20918 ⎘
Medicinal preparations containing peptides; Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
Sub-classes:COMPOSITIONS AND METHODS FOR THE TREATMENT OF LEUKODYSTROPHY AND WHOLE ANIMAL AND CELLULAR MODELS FOR IDENTIFYING EFFICACIOUS AGENTS FOR TREATMENT OF THE SAME
#2ALTERING INFLAMMATORY STATES OF IMMUNE CELLS IN VIVO BY MODULATING CELLULAR ACTIVATION STATES
#3ISCHEMIA/REPERFUSION INJURY
#4COMBINATION THERAPY FOR THE TREATMENT OF CANCER
#5Nutritional composition, a preparation method therefor, and uses thereof
#6TREATMENT FOR GINGIVITIS
#7REELIN COMPOSITIONS FOR TREATMENT OF NEUROLOGICAL DISORDERS
#8Composition and Use Method Therefor
#9PHARMACEUTICAL COMPOSITION COMPRISING RUNX3 GENE OR PROTEIN AS ACTIVE INGREDIENT FOR PREVENTION OR TREATMENT OF K-RAS MUTANT LUNG CANCER
#10FINE-TUNING INFLAMMATION BY ALTERING 3'UTR LENGTH
#11METHODS OF INCREASING READTHROUGH OF A PREMATURE TERMINATION CODON
#12Composition, Method, And Use of Netrin-1 In Preserving the Bone Marrow Niche to Promote Stem Cell Health
#13METHODS FOR INCREASING TYPE I, III, AND V COLLAGEN IN AN ANIMAL
#14METHOD FOR ENHANCING TRANSFERRIN RECEPTOR-BASED TRANSCYTOSIS ACROSS THE BLOOD BRAIN BARRIER
#15Compositions and Methods for Delivering CFTR Polypeptides
#16HTT REPRESSORS AND USES THEREOF
#17GLYCOTARGETING THERAPEUTICS
#18COMPOSITIONS COMPRISING PROTEIN DISULFIDE ISOMERASE AND METHODS OF PRODUCTION AND USE THEREOF
#19Secretoglobins for Suppression of Antibody Responses
#20PARTIAL EPIGENETIC REPROGRAMMING FOR LIVER DISEASE TREATMENT
#21REJUVENATING THE AGED SKELETAL MICROENVIRONMENT TO REVERSE AGE-RELATED BONE LOSS
#22GENE THERAPY TREATMENT
#23COMPOSITIONS AND METHODS UTILIZING A NOVEL HUMAN FOXO3 ISOFORM
#24METHODS AND COMPOSITIONS FOR PREVENTING AND TREATING ATHEROSCLEROSIS AND RELATED DISEASES
#25ENGINEERING NON-CYTOTOXIC DELIVERY OF PROTEINS BY T CELLS VIA FUSION TO NPC2
#26METHOD OF PREVENTING AND/OR TREATING CANCER BY SMALL- MOLECULE PROTEIN
#27PRODUCTION OF RECOMBINANT LUBRICIN
#28USE OF A SMALL NATIVE PEPTIDE ACTIVATOR OF SERCA PUMP FOR TREATMENT OF HEART FAILURE AND OTHER DISORDERS CHARACTERIZED BY CYTOSOLIC CALCIUM OVERLOAD
#29PHARMACEUTICAL COMPOSITION CONTAINING CBFbeta-EXPRESSING VASCULAR SMOOTH MUSCLE CELLS OR CULTURE FLUID THEREOF AS ACTIVE INGREDIENT FOR PREVENTION OR TREATMENT OF AGE-RELATED DISEASES
#30GENE THERAPY FOR FOXG1 SYNDROME
#31COMPOSITIONS AND METHODS FOR ENHANCING WNT SIGNALING FOR TREATING CANCER
#32COMPOSITIONS AND METHODS FOR TREATING CANCER
#33System and Method for the Production, Formulation and Use of Conditioned Media, Cultured Cells and the Factors Included Therein
#34Method of Inhibiting Durotaxis and/or Treating Fibrosis
#35TREATMENT OF NERVOUS SYSTEM INJURY AND NEURODEGENERATIVE DISORDERS AND RELATED CONDITIONS
#36METHOD FOR ROBOTIC ASSISTED HEART TRANSPLANT
#37CD40L-SPECIFIC TN3-DERIVED SCAFFOLDS FOR THE TREATMENT AND PREVENTION OF SJÖGREN'S SYNDROME
#38LOCO-REGIONAL PERFUSION OF A KIDNEY
#39RETROGRADE CORONARY VENOUS OR SINUS ADMINISTRATION OF THERAPEUTICS
#40Nutritive Polypeptides and Formulations Thereof, and Methods of Production and Use Thereof
#41METHODS OF ALTERING BONE GROWTH BY ADMINISTRATION OF SOST OR WISE ANTAGONIST OR AGONIST
#42METHODS AND COMPOSITIONS OF TREATING RETINAL DEGENERATIVE DISEASES
#43COMPOSITIONS AND SYNERGISTIC METHODS FOR TREATING INFECTIONS
#44P21 Expressing Monocytes for Cancer Cell Therapy
#45CELLULAR REPROGRAMMING TO REVERSE AGING AND PROMOTE ORGAN AND TISSUE REGENERATION
#46METHOD FOR PRODUCING NONHUMAN PRIMATE ANIMAL MODEL OF CEREBRAL INFARCTION AND PHARMACEUTICAL COMPOSITION FOR TREATMENT OF CEREBRAL INFARCTION
#47MATERIALS AND METHODS FOR TREATING FRIEDREICH'S ATAXIA
#48EPIGENETIC MODULATION OF GENOMIC TARGETS TO CONTROL EXPRESSION OF PWS-ASSOCIATED GENES
#49COMPOSITIONS AND METHODS FOR TREATING SKIN DISEASES, DISORDERS, AND CONDITIONS
#50HEMOPEXIN FORMULATIONS
#51ENHANCEMENT OF PHAGOCYTOSIS
#52NOVEL AAV3B CAPSID VARIANTS WITH ENHANCED HEPATOCYTE TROPISM
#53COMPOSITIONS FOR DRINKING WATER
#54IL-2 SUPERAGONISTS IN COMBINATION WITH ANTI-PD-1 ANTIBODIES
#55SLC26A4 REGULATORY ELEMENTS AND USES THEREOF
#56ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#57EPICARDIAL-DERIVED PARACRINE FACTORS FOR REPAIRING CARDIAC TISSUE
#58METHODS AND DEVICES FOR PROMOTING NERVE GROWTH AND REGENERATION
#59METHODS AND COMPOSITIONS FOR TUSC2 IMMUNOTHERAPY
#60ANTI-SYNUCLEINOPATHY PEPTIDE AND METHODS TO TREAT NEURODEGENERATIVE DISEASES
#61Compositions and Methods for Inhibiting T Cell Exhaustion
#62COMPOSITIONS AND METHODS FOR TREATING NON-AGE-ASSOCIATED HEARING IMPAIRMENT IN A HUMAN SUBJECT
#63DAIRY PRODUCT AND PROCESS
#64Adeno-Associated Virus Variant Capsids with Improved Lung Tropism and Uses Thereof
#65CELLULAR REPROGRAMMING TO REVERSE AGING AND PROMOTE ORGAN AND TISSUE REGENERATION
#66BAG3 METHODS AND USES FOR TREATMENT OF INFLAMMATION
#67A BIOENGINEERED AAV9 VECTOR CARRYING OPTIMIZED TRANSGENE FOR DUCHENNE MUSCULAR DYSTROPHY GENE THERAPY AND METHOD THEREOF
#68GENE THERAPY FOR FAM161A-ASSOCIATED RETINOPATHIES AND OTHER CILIOPATHIES
#69SMALL ACTIVATING RNA (saRNA) CAPABLE OF ACTIVATING CCAAT ENHANCER BINDING PROTEIN ALPHA (CEBPA) GENE, AND DELIVERY SYSTEM AND USE THEREOF
#70METHODS AND COMPOSITIONS FOR TREATING INFLAMMATORY AND AUTOIMMUNE CONDITIONS WITH ECM-AFFINITY PEPTIDES LINKED TO ANTI-INFLAMMATORY AGENTS
#71COMPOSITIONS AND METHODS FOR ANTIGEN-SPECIFIC TOLERANCE
#72USE OF CELL MEMBRANE-BOUND SIGNALING FACTORS
#73METHODS AND COMPOSITIONS FOR IMMUNOMODULATION
#74HETEROCYCLES AND USES THEREOF
#75COMPOSITIONS AND METHODS OF USE FOR THE TREATMENT OF DIABETES
#76METHODS FOR AFFECTING TISSUE-RESIDENT T CELLS
#77mRNA LIPID NANOPARTICLES FOR THE TREATMENT OF NIEMANN-PICK TYPE C DISEASE
#78COMPOSITIONS AND METHODS FOR EXPRESSING OTOFERLIN
#79VECTOR-BASED GENE THERAPY FOR ELONGATOR ACETYLTRANSFERASE COMPLEX SUBUNIT 1 (ELP1)
#80COMPOSITIONS COMPRISING PEDF-DERIVED SHORT PEPTIDES FOR THE TREATMENT OF DRY EYE DISEASES
#81METHODS FOR TREATING ACUTE CONDITIONS USING LIPID BINDING PROTEIN-BASED COMPLEXES
#82Modification and Compositions of Human Secretoglobin Proteins
#83METHOD FOR TREATMENT OF MYOTONIC DYSTROPHY COMBINING PROTEIN EXPRESSION AND RNA INTERFERENCE VECTOR DELIVERY WITH TISSUE DETARGETING
#84TRANSDERMAL DELIVERY DEVICE FOR PEPTIDE DELIVERY AND METHODS OF USE
#85NANOLIPOSOME COMPOSITIONS AND METHODS OF USING THE SAME
#86PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA
#87TREATMENT OF INFLAMMATORY CONDITIONS BY DELIVERY OF INTERLEUKIN-1 RECEPTOR ANTAGONIST FUSION PROTEIN
#88ISOFORM NELL-1 PEPTIDE
#89ANNEXIN A1 LIQUID PHARMACEUTICAL COMPOSITION
#90COMPOSITIONS AND METHODS FOR THE TREATMENT OF SEPSIS
#91Dry Powder Formulations for Messenger RNA
#92PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA
#93COMPOSITIONS AND METHODS FOR NUCLEIC ACID TRANSFER
#94GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING LOSS
#95COMPOSITIONS AND METHODS FOR TREATING CANCER BY INCREASING EXPRESSION OF OBSCN-AS1 LONG-NONCODING RNA
#96MONOMERIC ANNEXIN A5 FOR USE IN THE TREATMENT OF MACULAR OEDEMA OR RETINAL VEIN OCCLUSION
#97FUNCTIONAL POROSOME MANIPULATION
#98CELL CONVERSION
#99COMBINATION THERAPY FOR CLASSIC HODKIN'S LYMPHOMA
#100CONTROLLED EXPRESSION OF THERAPEUTICALLY RELEVANT BIOMOLECULES FOR LUMEN-LOCALIZED PAYLOADS IN BIOMIMETIC NANOVESICLES AND EXOSOMES
#101MATERIALS AND METHODS FOR TARGETING REGULATORY T CELLS FOR ENHANCING IMMUNE SURVEILLANCE
#102TREATMENT OF DISEASES RELATED TO COLONY-STIMULATING FACTOR 1 RECEPTOR DYSFUNCTION USING TREM2 AGONISTS
#103Compositions of Phosphorylated Tau Peptides and Uses Thereof
#104REVERSING AGING OF THE CENTRAL NERVOUS SYSTEM
#105TREATMENT OF NOCICEPTIVE PAIN
#106POWDERS CONTAINING A BUFFER SALT AND AN AMINO ACID, RECONSTITUTION OF SUCH A POWDER INTO A NUTRITIONAL PRODUCT, AND METHODS OF USING SUCH A NUTRITIONAL PRODUCT
#107RAAV VECTOR FOR THE TREATMENT OF COX20 DEFICIENCY
#108TREATMENTS FOR AGE-RELATED CELLULAR DYSFUNCTION
#109NOVEL METHODS AND COMPOSITION OF AAV VECTORS FOR THE TREATMENT OF FRIEDREICH'S ATAXIA
#110COMPOSITIONS FOR RESTORING MECP2 GENE FUNCTION AND METHODS OF USE THEREOF
#111RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR FOR TREATMENT OF IRON-ACCUMULATING NEURODEGENERATIVE DISEASES
#112DAP12 CONSTRUCTS AND THEIR USE TO ENHANCE DC VACCINES AND IMMUNOTHERAPIES
#113METHOD
#114LIPOPROTEIN COMPLEXES AND MANUFACTURING AND USES THEREOF
#115COMPOSITIONS AND METHODS FOR TREATING NON-AGE-ASSOCIATED HEARING IMPAIRMENT IN A HUMAN SUBJECT
#116METHOD FOR CONSTRUCTING HOTSPOT-DERIVED PEPTIDE-NUCLEIC ACID HYBRID MOLECULES ON BASIS OF IN VITRO SELECTION
#117REPROGRAMMED FUNCTIONAL FRAGMENT OF RECOMBINANT ONCOLYTIC VIRUS, COMBINATION, AND APPLICATION THEREOF
#118DEFORMABLE NANO-SCALE VEHICLES (DNVS) FOR TRANS-BLOOD BRAIN BARRIER, TRANS-MUCOSAL, AND TRANSDERMAL DRUG DELIVERY
#119LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF
#120Gene Therapy For Neurodegenerative Disorders
#121ENGINEERED SIRPá VARIANTS AND METHODS OF USE THEREOF
#122COMPOSITION FOR INDUCING REVERSE-AGING CONTAINING SLIT2 AND METHOD FOR INDUCING REVERSE-AGING
#123MICRO-DYSTROPHIN FOR HEART PROTECTION
#124PEG LIPIDOID COMPOUNDS
#125TREATMENT OF DISEASES RELATED TO ATP-BINDING CASSETTE TRANSPORTER 1 DYSFUNCTION USING TREM2 AGONISTS
#126METHOD AND COMPOSITIONS FOR NEURONAL REPROGRAMMING
#127Methods of Treating Retinal Degenerative Diseases Using AIMP2-DX2 and Optionally a Target Sequence for miR-142 and Compositions Thereof
#128METHODS AND COMPOSITIONS FOR DETOXIFICATION OF CHRONIC EXPOSURE TO TOXINS
#129SQSTM1 AND ITS USE IN CANCER THERAPY
#130METHODS AND COMPOSITIONS FOR TREATING INFLAMMATORY CONDITIONS ASSOCIATED WITH INFECTIOUS DISEASE
#131POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF
#132SYNERGISTIC COMBINATION OF RDCFV2 AND RDCVF2L FOR THE TREATMENT OF TAUOPATHIES
#133HISTATIN COMBINATIONS AND METHODS FOR TREATING OR INHIBITING CELL LOSS
#134METHODS OF TREATING FRIEDREICH'S ATAXIA
#135COMPOSITION FOR THE INHIBITION OF NRF2 AND USES THEREOF IN CANCER THERAPY
#136PTEROSTILBENE AND SILIBININ FOR PREVENTING, AMELIORATING OR REDUCING RADIATION-INDUCED DISEASES
#137B-CELL LYMPHOMA 2-ASSOCIATED ANTHANOGENE 3 (BAG3) GENE THERAPY USING AAV VECTOR
#138HUMAN EPENDYMA-SPECIFIC PROMOTER AND USES THEREOF
#139THERAPEUTIC LAMA2 PAYLOAD FOR TREATMENT OF CONGENITAL MUSCULAR DYSTROPHY
#140METHODS AND COMPOSITIONS FOR MODULATION OF TAU PROTEINS
#141METHOD OF TREATING, AMELIORATING AND/OR PREVENTING POLYCYSTIC KIDNEY DISEASE
#142PHARMACEUTICAL USE OF FAM19A5 INVOLVED IN REGULATING GLIOGENESIS
#143METHOD FOR PREVENTING OR TREATING CANCER BY BLOCKING EXCESSIVE PRODUCTION OF PHOSPHORYLATED VIMENTIN
#144ICE-BASED LIPID NANOPARTICLE FORMULATIONS FOR DELIVERY OF MRNA
#145METHODS FOR TREATING LEUKOCYTOSIS, ENDOTHELIAL DYSFUNCTION AND CARDITIS USING LIPID BINDING PROTEIN-BASED COMPLEXES
#146LYOPHILIZED LIPID NANOPARTICLES AND METHODS OF THEIR USE
#147CAPSIDS FOR PLAKOPHILLIN-2 GENE THERAPY
#148TRANSLATION ENHANCING NUCLEIC ACID COMPOUNDS: ASO COUPLED TRANSLATION – UPREGULATION 1 (ACT-UP1) AND USES THEREOF
#149PLAKOPHILLIN-2 GENE THERAPY TREATMENT METHODS
#150ACTRII PROTEINS FOR THE TREATMENT OF PULMONARY ARTERIAL HYPERTENSION (PAH)
#151ENGRAFTMENT OF STEM CELLS WITH A COMBINATION OF AN AGENT THAT TARGETS STEM CELLS AND MODULATION OF IMMUNOREGULATORY SIGNALING
#152METHODS OF MODULATING PROGRANULIN EXPRESSION USING ANTISENSE OLIGONUCLEOTIDES TARGETING REGULATORY RNAS
#153COMPOSITIONS AND METHODS FOR TREATING SENSORINEURAL HEARING LOSS, VESTIBULAR DYSFUNCTION AND VISION LOSS USING PROTOCADHERIN 15 DUAL VECTOR SYSTEMS
#154RECOMBINANT THERAPEUTIC FMR1 CONSTRUCTS AND METHODS OF TREATING FRAGILE X SYNDROME AND RELATED DISORDERS
#155HEPARIN-ASSOCIATED POLYPEPTIDES AND USES THEREOF
#156NANOLIPOSOME COMPOSITIONS AND METHODS OF TREATING STROKE
#157TARGETTING ACTIVITY OF THE MITF FAMILY AS A THERAPEUTIC FOR REGULATING GENE EXPRESSION NETWORKS IMPLICATED IN B CELL HOMEOSTASIS, GERMINAL CENTER RESPONSES, AND TOLERANCE
#158NON-OPIOID METHODS FOR TREATING PAIN
#159THERAPEUTIC AND DIAGNOSTIC METHODS AND COMPOSITIONS FOR NEURODEGENERATIVE DISEASES
#160PERMANENT EPIGENETIC GENE SILENCING
#161METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
#162CARDIO-PROTECTIVE EFFECT OF VASOCONSTRICTION-INHIBITING FACTOR (VIF)
#163Compositions and Methods for Treating Striatonigral Degeneration
#164DAIRY PRODUCT AND PROCESS
#165GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING LOSS
#166ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RETINAL REGIONS
#167Treatment for Ocular Fibrosis
#168PROCESSES FOR MAKING AND USING A MESENCHYME STEM CELL SECRETOME FOR LIMBAL STEM CELL DEFICIENCY (LSCD) TREATMENT
#169POLYNUCLEOTIDES ENCODING FANCONI ANEMIA, COMPLEMENTATION GROUP PROTEINS FOR THE TREATMENT OF FANCONI ANEMIA
#170Cochlear and/or vestibular cell specific promoter and use thereof
#171ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL GANGLION CELLS AND/OR RETINAL PIGMENT EPITHELIUM CELLS
#172USE OF BOVINE SPLEEN PEPTIDE POWDER IN IMPROVING SLEEP, PREVENTING OR TREATING DEPRESSION, OR IMPROVING INTESTINAL FUNCTION
#173COMPOSITIONS AND METHODS
#174Method of Treating Osteoarthritis
#175CONSTRUCTS, VIRAL VECTORS AND PHARMACEUTICAL COMPOSITIONS COMPRISING LONG NONCODING RNA ANRIL FOR TREATMENT OF DISEASE
#176PHYTOECDYSONES AND/OR 20-HYDROXYECDYSONE DERIVATIVES IN COMBINATION WITH AN ACTIVE INGREDIENT FOR RESTORING SMN EXPRESSION, FOR USE IN THE TREATMENT OF SPINAL MUSCULAR ATROPHY
#177ACTIVIN RECEPTOR TYPE IIB VARIANTS AND METHODS OF USE THEREOF
#178Intrathecal Delivery of Recombinant Adeno-Associated Virus 9
#179METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY WITH A VIRAL VECTOR
#180DRUG AND METHOD FOR FORMING GABAERGIC NEURONS
#181Unknown
#182USE OF FOLLISTATIN-LIKE 1 (FSTL1) IN CARDIOMETABOLIC HEART FAILURE
#183SYSTEMS, METHODS, AND COMPOSITIONS FOR RESCUING PROTEIN MISFOLDING
#184CD300LD INHIBITOR AND USE THEREOF IN THE PREPARATION OF TUMOR IMMUNOTHERAPY PRODUCTS
#185NUTRITIONAL COMPOSITION
#186PROCESSES FOR MAKING AND USING A CELLULAR FIBRONECTIN COMPOSITION
#187NATURAL TISSUE SCAFFOLDS AS TISSUE FILLERS
#188METHODS FOR REGULATING FREE FATTY ACID FLUX USING FAT SPECIFIC PROTEIN 27 (FSP27) COMPOSITIONS
#189USE OF ANNEXINS IN PREVENTING AND TREATING CARDIAC NEURONAL CELL MEMBRANE INJURY AND DISEASE
#190PHOSPHORYLATION OF P53 AS A PROGNOSTIC OR DIAGNOSTIC MARKER FOR THE TREATMENT OF SENESCENT CELLS IN A MAMMAL
#191METHODS FOR NEURAL REGENERATION IN VIVO AND USES THEREOF
#192Compositions and Methods for Diagnosing and Treating Intellectual Disabilities
#193Compositions and Methods to Prevent, Inhibit or Treat Autoimmune and Vascular Disease
#194RECOMBINANT PROTEIN FOR ULCERATIVE COLITIS TREATMENT OR PREVENTION AND COMPOSITION FOR ULCERATIVE COLITIS TREATMENT OR PREVENTION CONTAINING THE SAME
#195HUMAN UMBILICAL CORD COMPOSITION FOR TREATMENT OF PEYRONIE'S DISEASE
#196Materials & Methods for Treatment of Macular Degeneration
#197LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF
#198SCO-spondin-derived polypeptides for enhancing synaptic transmission
#199Antisecretory Factor for Use in Treatment and/or Prevention of Acute Respiratory Failure
#200HIF-1 ACTIVATORS AND USES THEREOF
#201PERITONEAL DIALYSIS FLUID COMPOSITION COMPRISING A COMPLEMENT INHIBITOR
#202THERAPEUTIC FACTORS FOR THE TREATMENT OF POLYQ DISEASES
#203C-TYPE NATRIURETIC PEPTIDE VARIANTS TO TREAT SKELETAL DYSPLASIA IN CHILDREN
#204COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS) AND RELATED DISORDERS
#205SYNERGISTIC COMPOSITIONS FOR IMPROVING MINERAL BIOACCESSIBILITY
#206TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS
#207DRY POWDER INHALER AND SYSTEM FOR DRUG DELIVERY
#208METHODS OF GENERATING A POPULATION OF NEURONS FROM HUMAN GLIAL PROGENITOR CELLS AND GENETIC CONSTRUCTS FOR CARRYING OUT SUCH METHODS
#209ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#210COMPOSITIONS AND METHODS FOR TREATING DISEASE
#211METHODS AND PHARMACEUTICAL COMPOSITIONS FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY ASSOCIATED WITH FRIEDREICH ATAXIA
#212PEPTIDIC INHIBITORS OF AMYLOID SELF- AND CROSS-ASSEMBLY
#213Medical application and pharmaceutical composition of UbV.E4B protein
#214PREVENTING ALU SINES-MEDIATED PATHOLOGIES
#215LUTEIN FOR USE IN INHIBITING MAST CELL DEGRANULATION
#216DRY POWDER INHALER AND SYSTEM FOR DRUG DELIVERY
#217DRY POWDER INHALER AND SYSTEM FOR DRUG DELIVERY
#218HYDRODYNAMIC GENE DELIVERY
#219COMPLEXES FOR TREATING SENSITIVITY
#220Mutant Peptides And Methods Of Treating Subjects Using The Same
#221COMPOSITIONS AND METHODS FOR TREATING METABOLIC DISORDERS
#222COMPOSITION FOR PREVENTION OR TREATMENT OF DRY EYE DISEASE COMPRISING HAPLN1
#223UTERINE CANCER TREATMENTS
#224METHODS USING SURFACE-EXPRESSIBLE ACTIVATABLE EPITOPES TO LOCALIZE AND/OR TREAT DISEASED CELLS
#225TREATMENT OF ACQUIRED FOCAL EPILEPSY
#226DISRUPTION OF THE SECRETION OF INSULIN-LIKE GROWTH FACTOR 2 FOR CANCER TREATMENT
#227NOVEL PEPTIDES AND COMBINATION OF PEPTIDES FOR USE IN IMMUNOTHERAPY AGAINST BREAST CANCER AND OTHER CANCERS
#228COMPOSITIONS AND METHODS FOR TREATING CENTRAL NERVOUS SYSTEM INJURY
#229METHODS AND COMPOSITIONS FOR TREATING DRY EYE, TEAR HYPEROSMOLARITY-INDUCED PATHOLOGICAL CHANGES, AND OTHER OCULAR CONDITIONS
#230MODIFIED EXTRACELLULAR VESICLES THAT SPECIFICALLY TARGET KIDNEYS AND METHODS OF PREPARATION AND APPLICATIONS THEREOF
#231METHODS AND COMPOSITIONS FOR DETERMINING RISK OF AUTISM SPECTRUM DISORDERS
#232TRIPLE COMBINATION ANTIBODY THERAPIES
#233ANTICONVULSANT AND NEUROPROTECTIVE AGENT
#234RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT SYNDROME AND RELATED DISORDERS
#235ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF
#236MRNA REGULON THERAPY FOR THE TREATMENT OF HAPLOINSUFFICIENCY DISORDERS
#237TARGETED OESOPHAGEAL ADMINISTRATION OF ZN-ALPHA2-GLYCOPROTEINS (ZAG), METHODS AND FORMULATIONS THEREOF
#238THERAPEUTIC PEPTIDES
#239COMPOSITIONS AND METHODS FOR TREATING DISEASE
#240GJB2 REGULATORY ELEMENTS AND USES THEREOF
#241GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING STATHMIN 2 (STMN2) AND USES THEREOF
#242POLYPEPTIDES FOR TREATMENT OF CANCER
#243CYTOKINE MODULATION
#244METHODS AND COMPOSITIONS FOR INHIBITING FIBROSIS AND SCARRING
#245TREATMENT OF VAGINAL DYSBIOTIC CONDITIONS WITH ASSOCIATED ELEVATED VAGINAL CALPROTECTIN
#246PRODRUG COMPRISING A DRUG-LINKER CONJUGATE
#247USE OF LINK-TSG6 FOR THE TREATMENT OF OSTEOARTHRITIC PAIN
#248GENE THERAPY FOR GENETIC HEARING LOSS
#249POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF
#250WHEY PROTEIN MICELLES AGAINST MUSCLE ATROPHY AND SARCOPENIA
#251COMPOUND, COMPOSITION AND METHODS FOR LOWERING CIRCULATING GLUCOSE
#252METHODS AND COMPOSITIONS RELATING TO CHONDRISOMES FROM BLOOD PRODUCTS
#253TWO-PRONGED TREATMENT FOR NIEMANN PICK TYPE C DISEASE
#254COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEASES AND NEUROGENERATIVE DISORDERS
#255BRAIN-METASTATIC LUNG CANCER CELL LINE AND USE OF NOGGIN AS MARKER FOR BRAIN METASTASIS OF LUNG CANCER
#256METHOD FOR MODULATING APPETITE
#257CIRCULAR RNA VACCINES AND METHODS OF USE THEREOF
#258TRIGGER NUCLEIC ACIDS AND RNA-BINDING PROTEINS FOR UPREGULATING GENE EXPRESSION
#259METHODS AND COMPOSITIONS FOR TREATING DIABETES, AND METHODS FOR ENRICHING MRNA CODING FOR SECRETED PROTEINS
#260COMPOSITIONS AND METHODS FOR TREATING CANCER
#261MODIFIED ADENO-ASSOCIATED VIRUS VECTOR
#262GENERATION OF LARGE PROTEINS BY CO-DELIVERY OF MULTIPLE VECTORS
#263Compositions And Methods For Regulating ZNF865
#264MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA
#265COMPOSITION AND METHODS FOR MODULATION OF ELOVL2
#266METHODS AND COMPOSITIONS FOR REGENERATING HAIR CELLS AND/OR SUPPORTING CELLS
#267METHODS OF TREATING NEURODEGENERATIVE DISEASES
#268Reconstituted HDL Formulation
#269COMPOSITIONS AND METHODS FOR TREATING CANCER
#270DRY POWDER INHALER AND SYSTEM FOR DRUG DELIVERY
#271METHODS AND SYSTEMS FOR CORRECTING MUTATIONS IN PRPH2
#272ENGINEERED MUSCLE TARGETING COMPOSITIONS
#273USE OF PBX1 IN PROMOTING HAIR GROWTH
#274ALLEVIATING DRUG NEPHROTOXICITY
#275CARD9 ATTENUATES AB PATHOLOGY AND MODIFIES MICROGLIAL RESPONSES IN AN ALZHEIMER’S DISEASE
#276COMPOSITIONS AND METHODS FOR PREVENTION AND TREATMENT OF GENETIC DISEASE
#277ACTRII PROTEINS FOR THE TREATMENT OF PULMONARY ARTERIAL HYPERTENSION (PAH)
#278COMPOSITIONS AND METHODS FOR ENHANCING CARDIOMYOCYTE TRANSPLANT ENGRAFTMENT
#279PHARMACEUTICAL COMPOSITION FOR PREVENTION OR TREATMENT OF INFLAMMATORY DISEASE OR PAIN, COMPRISING MESENCHYMAL STEM CELLS EXPRESSING PTX-3, TIMP1 AND BDNF AS ACTIVE INGREDIENT
#280IMMUNOTHERAPY AGAINST SEVERAL TUMORS INCLUDING LUNG CANCER
#281GENE THERAPY METHODS FOR TREATMENT OF DIABETES
#282ENDOGENOUS GENE REGULATION TO TREAT NEUROLOGICAL DISORDERS AND DISEASES
#283HOST PROTEASES ESSENTIAL FOR PARAINFLUENZA SPREAD IN THE HUMAN LUNG: POTENTIAL TARGETS FOR ANTIVIRAL INTERVENTIONS
#284Use Of Liposomes To Deliver A Protein And A Gene Encoding The Protein To A Live Cell
#285Compositions and Methods for Gene Delivery to the Airways and/or Lungs
#286PROTEINS WITH CARDIOPROTECTIVE ACTIVITY
#287METHODS AND COMPOSITIONS FOR IMPROVED MOLECULAR THERAPIES OF MULTIGENIC DISEASES
#288COMPOSITION AND METHODS FOR TREATING RADIATION INDUCED INJURY
#289TREATMENT OF AGE-RELATED MACULAR DEGENERATION
#290COMPOSITIONS, METHODS AND USES OF MESSENGER RNA
#291NOVEL IMMUNOTHERAPY AGAINST SEVERAL TUMORS INCLUDING GASTROINTESTINAL AND GASTRIC CANCER
#292HYALURONIC ACID BINDING PEPTIDE AS A THERAPEUTIC TO CONTROL FIBROBLAST ACTIVATION AND FIBROTIC CAPSULE FORMATION
#293BLOCKING AND REVERSING EXTRACELLULAR VESICLE DRIVEN TRANSCRIPTOMIC TRANSFORMATION WITH ANNEXIN V TREATMENT
#294FUSED IN SARCOMA (FUS) NUCLEAR TRANSLOCATION INHIBITORS FOR PREVENTING FIBROSIS
#295METHODS AND COMPOSITIONS FOR TREATING BAG-3 RELATED CARDIOMYOPATHY WITH A VIRAL VECTOR
#296POLYPEPTIDE SEQUENCE OF KDM6B AND APPLICATION OF KDM6B IN REGULATING AND CONTROLLING FUNCTION OF MESENCHYMAL STEM CELL
#297THERAPEUTIC AGENT FOR REFRACTORY VIRAL INFECTIONS
#298DIAGNOSTIC AND THERAPEUTIC METHODS USING HEME AS A BIOMARKER FOR CELLULAR AND TISSUE DAMAGE
#299IMMUNOGLOBULINS AND USES THEREOF
#300HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS