21025 ⎘
Medicinal preparations containing peptides; Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof; Enzymes; Proenzymes; Derivatives thereof Transferases (2)
MEDICINAL PREPARATION FOR COMBINED GENE-DIRECTED ENZYME PRODRUG THERAPY AND IMMUNOTHERAPY OF SOLID MALIGNANT TUMOURS (EMBODIMENTS)
#2ALTERING INFLAMMATORY STATES OF IMMUNE CELLS IN VIVO BY MODULATING CELLULAR ACTIVATION STATES
#3GENE THERAPY FOR DISEASES CAUSED BY UNBALANCED NUCLEOTIDE POOLS INCLUDING MITOCHONDRIAL DNA DEPLETION SYNDROMES
#4HYBRID AAV VECTOR ENHANCING TRANSGENE EXPRESSION IN THE LIVER
#5FIBROBLAST CELL THERAPY FOR TREATMENT OF OSTEOPOROSIS
#6Compositions and Methods for Treating Disorders Associated with Cone Photoreceptor Cells
#7GENE THERAPY FOR OCULAR DISEASE
#8METHODS FOR IMPROVED THERAPEUTIC USE OF RECOMBINANT AAV
#9METHODS OF TREATING CANCERS
#10CELLULAR COMPOSITIONS AND METHODS OF TREATMENT I
#11PROTEIN OR POLYPEPTIDE-LOADED EXTRACELLULAR VESICLE DELIVERY PLATFORM AND APPLICATION THEREOF
#12REGULATION OF RAN TRANSLATION BY PKR AND EIF2A-P PATHWAYS
#13METHODS AND SYSTEMS FOR IMPROVED NUCLEIC ACID DELIVERY VIA ULTRASOUND
#14PROTEIN SCAFFOLDS FOR DISORDERED REGIONS
#15COMPOSITIONS AND METHODS FOR MODULATING CHOLESTEROL EFFLUX
#16Use Of P55gamma As Therapeutic Target For Aortic Dissection (ad)
#17TREATING CHRONIC INFLAMMATION AND CANCER BY MACROPHAGE POLARIZATION
#18COMPOSITIONS AND METHODS FOR COMPARTMENT-SPECIFIC CARGO DELIVERY
#19Nutritive Polypeptides and Formulations Thereof, and Methods of Production and Use Thereof
#20Hyperactive variants of the transposase protein of the transposon system Sleeping Beauty
#21SELECTIVE FUNCTIONAL ENHANCEMENT OF STEM CELLS AND OR THEIR GENETIC MATERIAL, WITH GENE TRANSFECTION FOR SHORT-AND LONG-TERM TREATMENT OF AGE-RELATED DISEASE STATES
#22SECRETED RNA THERAPEUTICS FOR NUCLEAR DELIVERY
#23IMMUNOMODULATORY COMPOSITIONS AND METHODS
#24Methods of Administering 3,4-Diaminopyridine
#25NANOPARTICLE COMPLEXES FOR ENHANCED SAFETY
#26ALZHEIMER'S DISEASE GENE THERAPEUTICS AND METHODS OF USE THEREOF
#27COMPOSITIONS AND METHODS FOR TREATING BACTERIAL DISEASE
#28AAV GENE THERAPY FOR TREATING A NERVOUS SYSTEM DISEASE
#29METHODS TO TREAT ACUTE KIDNEY INJURY WITH A FLUID
#30PROTEIN SCAFFOLDS FOR DISORDERED REGIONS
#31KYNURENINE AMINOTRANSFERASE AND PRODUCTS THEREOF FOR THE TREATMENT OF ARTHRITIC DISEASES
#32CANCER IMMUNOTHERAPIES TO PROMOTE HYPERACUTE REJECTION
#33Dry Powder Formulations for Messenger RNA
#34TRINUCLEOTIDE CAP ANALOGS, PREPARATION AND USES THEREOF
#35ALK POLYPEPTIDES AND METHODS OF USE THEREOF
#36COMPOSITIONS FOR AND METHODS OF TREATING AND/OR PREVENTING GLYCOGEN STORAGE DISEASE TYPE VI AND TYPE IX
#37MULTIPARTITE RECEPTOR AND SIGNALING COMPLEXES
#38COMPOSITIONS AND METHODS FOR FACILITATING DELIVERY OF SYNTHETIC NUCLEIC ACIDS TO CELLS
#39METHOD FOR EXPRESSING A MUSCLE-SPECIFIC GENE AND CASSETTES FOR SAME
#40TREATMENT OF MUSCLE FIBROSIS
#41REDUCING THE RISK OF MAJOR ADVERSE CARDIAC EVENTS
#42REDUCING THE RISK OF MAJOR ADVERSE CARDIAC EVENTS
#43METHODS OF USING LONG NON-CODING RNA-8 (TROLL-8) AS A TARGET FOR CANCER DETECTION AND TREATMENT
#44VARIANTS OF THE HUMAN ATM PROTEIN FOR THE TREATMENT OF DISEASES RELATED TO AT LEAST ONE MUTATION OF THE ATM GENE
#45PEG LIPIDOID COMPOUNDS
#46METHODS OF TREATING DISEASES ASSOCIATED WITH TRAUMATIC BRAIN INJURY
#47Gene Therapy for NMNAT1-Associated Retinal Degeneration
#48CHOLIX TOXIN-DERIVED FUSION MOLECULES FOR ORAL DELIVERY OF BIOLOGICALLY ACTIVE CARGO
#49LYOPHILIZED LIPID NANOPARTICLES AND METHODS OF THEIR USE
#50PROCESS FOR THE PREPARATION OF ERYTHROCYTES LOADED WITH ONE OR MORE SUBSTANCES OF PHARMACEUTICAL INTEREST AND SO OBTAINED ERYTHROCYTES
#51NAMPT FOR WOUND-HEALING AND STIMULATING HAIR GROWTH AND/OR REGROWTH
#52COMPOSITIONS AND METHODS FOR TREATING PULMONARY HYPERTENSION
#53LIQUID-DISPERSIBLE HALOPYRUVATE FORMULATIONS AND ASSOCIATED METHODS
#54COMPOSITIONS AND METHODS FOR TREATING PULMONARY HYPERTENSION
#55PERMANENT EPIGENETIC GENE SILENCING
#56CHIMERIC IL-10/CARRIER CONSTRUCTS FOR TREATMENT OF POUCHITIS AND METHODS OF USE
#57USE OF p55gamma PROTEIN OR ENCODING GENE THEREOF AS TARGET IN PREPARATION OF DRUG FOR PREVENTING AND/OR TREATING VASCULAR CALCIFICATION
#58METHODS TO TREAT, PREVENT, OR REDUCE HYPERAMMONEMIA
#59CGAS SUPER-ENZYMES FOR CANCER IMMUNOTHERAPY
#60Viral Vectors For Treating Neurogenic Detrusor Overactivity
#61METHODS AND PRODUCTS FOR NUCLEIC ACID PRODUCTION AND DELIVERY
#62LIPID NANOPARTICLES FOR TARGETED DELIVERY OF MRNA
#63COMPOSITIONS AND METHODS FOR TREATING AND/OR PREVENTING GLYCOGEN STORAGE DISEASES
#64TARGET SUBSTRATE PROTEIN DEGRADATION PLATFORM
#65LIPID NANOPARTICLES FOR DELIVERY TO THE EYE OR EAR
#66A DRUG FOR USE IN THE TREATMENT OF MUSCLE SPASTICITY BY CHEMICAL MUSCLE DENERVATION
#67METHODS OF CYTOTOXIC GENE THERAPY TO TREAT TUMORS
#68COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#69ENGINEERED PROBIOTICS AND THE APPLICATIONS THEREOF
#70PREPARATION OF NOVEL TRITERPENE ALCOHOL DERIVATIVES WITH ENHANCED BIOAVAILABILITY FOR CANCER, INFLAMMATION AND PAIN TREATMENT
#71Lyophilized Pharmaceutical Compositions Comprising A Lipid Nanoparticle
#72PEPTIDES FOR TREATING PAIN OR REDUCING PAIN SENSITIVITY
#73COMPOSITION AND METHODS FOR TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#74IMMUNE SYSTEM MODULATORS AND USES THEREOF
#75COMPOSITIONS AND METHODS FOR TREATING INFECTIOUS DISEASES
#76COMPOSITIONS AND METHODS OF USING TWO-PROMOTER VECTOR FOR TREATMENT OF LYSOSOMAL STORAGE DISORDERS
#77INHIBITOR-RESISTANT MGMT MODIFICATIONS AND MODIFICATION OF MGMT-ENCODING NUCLEIC ACIDS
#78SINGLE-VECTOR GENE CONSTRUCT COMPRISING INSULIN AND GLUCOKINASE GENES
#79SMALL EXTRACELLULAR VESICLES EXPRESSING A DOMINANT NEGATIVE AMPK ALPHA 1 MUTANT FOR USE IN THE TREATMENT OF OBESITY
#80COMPOSITIONS AND METHODS FOR TREATING MITOCHONDRIAL NEUROGASTROINTESTINAL ENCEPHALOPATHY
#81CIRCULAR RNA VACCINES AND METHODS OF USE THEREOF
#82DEGRADATION OF TOXINS IN VIVO
#83COMPOSITIONS AND METHODS OF FAS INHIBITION
#84COMPOSITION AND METHODS FOR MODULATION OF ELOVL2
#85THIOESTER CATIONIC LIPIDS
#86m6A mRNA MODIFICATION IN CANCER TREATMENT
#87ENGINEERED MICROORGANISM FOR TREATING HYPERPHENYLALANINEMIA AND USE THEREOF
#88MITAPIVAT THERAPY AND MODULATORS OF CYTOCHROME P450
#89CHOLINE ACETYLTRANSFERASE AS A THERAPY FOR ENDOTOXEMIA, SEPSIS, COLITIS AND INFLAMMATORY DISEASES
#90POLYPEPTIDE SEQUENCE OF KDM6B AND APPLICATION OF KDM6B IN REGULATING AND CONTROLLING FUNCTION OF MESENCHYMAL STEM CELL
#91COMPOSITIONS AND METHODS FOR THE TREATMENT OF NONALCOHOLIC STEATOHEPATITIS (NASH) FIBROSIS
#92EUKARYOTIC ELONGATION FACTOR-2 KINASE AS A CYTOTOXIC T LYMPHOCYTES BOOSTER
#93METHODS AND MATERIALS FOR GALGT2 GENE THERAPY
#94MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF BIOLOGICS AND PROTEINS ASSOCIATED WITH HUMAN DISEASE
#95METHOD FOR DECREASING DEGENERATION OF RETINAL GANGLION CELLS
#96METHOD FOR TREATING AND/OR PREVENTING REGNASE-1-RELATED DISEASE
#97GENE THERAPY FOR GALACTOSEMIA
#98POLYPEPTIDE BASED ON RECEPTOR-INTERACTING PROTEIN KINASE-3 METHYLATION MODIFICATION AND APPLICATION THEREOF IN CELL NECROPTOSIS-RELATED DISEASES
#99AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GALACTOSIDASE AND THEIR USE TO TREAT FABRY DISEASE
#100USE OF LOW pH ACTIVE ALPHA-1,4;/1,6-GLYCOSIDE HYDROLASES (GLCH) AS A FEED ADDITIVE FOR RUMINANTS TO ENHANCE STARCH DIGESTION
#101KYNURENINE AMINOTRANSFERASE AND PRODUCTS THEREOF FOR THE TREATMENT OF INFLAMMATORY BOWEL DISEASES
#102Lyophilized Pharmaceutical Compositions Comprising a Lipid Nanoparticle
#103METHODS FOR THE TEMPORAL REGULATION OF REPROGRAMMING FACTORS IN MAMMALIAN CELLS
#104CATIONIC POLYMERS
#105ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METHODS OF USE AND MANUFACTURE
#106ASH1L degraders and methods of treatment therewith
#107ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METHODS OF USE AND MANUFACTURE
#108COMPOSITIONS COMPRISING A LECITHIN CHOLESTEROL ACYLTRANSFERASE VARIANT AND USES THEREOF
#109GENE THERAPY VECTORS FOR USE IN PARKINSON'S DISEASE
#110POST-TRANSLATIONAL MODIFICATION CHIMERIC MOLECULE
#111MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF PROTEINS ASSOCIATED WITH HUMAN DISEASE
#112GEL PRECURSOR COMPOSITION, METHOD FOR PRODUCING GEL, AND METHOD FOR ACTIVATING ENZYME
#113Inhibition of Diacylglycerol Kinase to Augment Adoptive T cell Transfer
#114Ligand Binding Molecules and Uses Thereof
#115COMPOSITION FOR IMPROVING, PREVENTING OR TREATING INFLAMMATORY BOWEL DISEASE COMPRISING NAMPT-DERIVED PEPTIDE AS ACTIVE INGREDIENT
#116NEUROPROTECTION GENE THERAPY
#117GNE AS A THERAPEUTIC AGENT
#118VARIANTS OF SIRT6 FOR USE IN PREVENTING AND/OR TREATING AGE-RELATED DISEASES
#119BISPECIFIC ANTIBODIES USING FUNCTIONALIZED POLY-ADP-RIBOSE POLYMERS
#120ASH1L INHIBITORS AND METHODS OF TREATMENT THEREWITH
#121NME INHIBITORS AND METHODS OF USING NME INHIBITORS
#122COMPOUNDS, COMPOSITIONS, METHODS, AND KITS RELATING TO TELOMERE EXTENSION
#123RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR LESCH-NYHAN DISORDERS AND USES THEREOF
#124RECOMBINANT AAV VECTORS EXPRESSING OSTEOPROTECTIVE GENES, INCLUDING HAS2 AND LUBRICIN, USEFUL IN THE TREATMENT OF OSTEOARTHRITIS AND RELATED JOINT CONDITIONS IN MAMMALS
#125COMPOSITIONS AND METHODS FOR ENHANCED PROTEIN PRODUCTION
#126DESIGNED CONSTITUTIVELY ACTIVE CYCLIC GMP-AMP SYNTHASE AS A GENETICALLY ENCODED STIMULANT OF INTERFERONS
#127Expression of Bacterial Dinucleotide Cyclases
#128Treatment Of B27-Negative Uveitis With Inositol Polyphosphate Multikinase (IPMK) Therapeutic Agents Or Indoleamine 2,3-dioxygenase 2 (IDO2) Agonists
#129TREATMENTS AND METHODS FOR TREATING ALZHEIMER'S DISEASE
#130Viral Vectors For Treating Neurogenic Detrusor Overactivity
#131USE OF PERTUSSIS TOXIN AS A THERAPEUTIC AGENT
#132CHOLIX TOXIN-DERIVED FUSION MOLECULES FOR ORAL DELIVERY OF BIOLOGICALLY ACTIVE CARGO
#133TREATMENT OF EYE DISEASES WITH FRUCTOSYL-AMINO ACID OXIDASE
#134COMPOSITIONS FOR TREATING HEART DISEASE BY INHIBITING THE ACTION OF mAKAP-beta
#135CHOLIX TOXIN-DERIVED FUSION MOLECULES FOR ORAL DELIVERY OF BIOLOGICALLY ACTIVE CARGO
#136METHODS OF TREATING ADENOCARCINOMA WITH HUMAN MICROBIOTA DERIVED N-ACYL AMIDES
#137A PHARMACEUTICALLY ACCEPTABLE AQUEOUS GEL COMPOSITION FOR MRNA DELIVERY
#138BACTERIA ENGINEERED TO TREAT DISORDERS IN WHICH OXALATE IS DETRIMENTAL
#139BIOMARKERS OF AGING FOR DETECTION AND TREATMENT OF DISORDERS
#140COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#141Application Of PI4KIIIA Protein And Related Membrane Protein Complex In Treating Alzheimer's Disease
#142CANCER THERAPY
#143METHODS AND COMPOSITIONS FOR REJUVENATING CNS GLIAL POPULATIONS BY SUPPRESION OF TRANSCRIPTION FACTORS
#144Treatment of Anthrax with Pegylated Capsule-Degrading Enzyme
#145MUC16 PROMOTER CONTAINING VIRUS
#146ANTI-INFLAMMATORY PEPTIDES AND COMPOSITION COMPRISING THE SAME
#147TGF-BETA SUPERFAMILY TYPE I AND TYPE II RECEPTOR HETEROMULTIMERS AND USES THEREOF
#148INHIBITORS OF CYTOCHROME P450 FAMILY 7 SUBFAMILY B MEMBER 1 (CYP7B1) FOR USE IN MOBILIZATION OF HEMATOPOIETIC STEM AND PROGENITOR CELLS
#149Viral Vectors For Treating Neurogenic Detrusor Overactivity
#150GENOME EDITING SYSTEMS COMPRISING REPAIR-MODULATING ENZYME MOLECULES AND METHODS OF THEIR USE
#151MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF CYTOPLASMIC AND CYTOSKELETAL PROTEINS
#152Use of pertussis toxin as a therapeutic agent
#153CHOLIX TOXIN-DERIVED FUSION MOLECULES FOR ORAL DELIVERY OF BIOLOGICALLY ACTIVE CARGO
#154Cancer Stem Cell Targeted Cancer Vaccines
#155COUPLING ENDONUCLEASES WITH END-PROCESSING ENZYMES DRIVES HIGH EFFICIENCY GENE DISRUPTION
#156NOVEL USE OF MPK38/MELK AS THERAPEUTIC AGENT FOR OBESITY OR METABOLIC DISEASES SPECIFIC TO MIDDLE-AGED MEN
#157Anti-inflammatory peptides and composition comprising the same
#158PROBIOTIC SULFATION OF SECONDARY BILE ACIDS
#159COMPOSITIONS AND METHODS FOR THE TREATMENT OF ISCHEMIA AND CARDIOMYOPATHY
#160TELOMERASE REVERSE TRANSCRIPTASE-BASED THERAPIES
#161THERAPEUTIC COMBINATIONS INCLUDING INHIBITORS OF THE P2X4 RECEPTOR FOR TREATING AND PREVENTING PROLIFERATIVE DISORDERS
#162Therapy for Mitochondrial Fatty Acid Beta-Oxidation and Transport Disorders
#163ACTIVATING MITOTIC CHECKPOINT CONTROL MECHANISMS
#164METHODS AND COMPOSITIONS
#165Process of Preparing mRNA-Loaded Lipid Nanoparticles
#166COMPOSITIONS FOR FACILITATING MEMBRANE FUSION AND USES THEREOF
#167LUNG TREATMENT COMPOSITIONS
#168MITAPIVAT THERAPY AND MODULATORS OF CYTOCHROME P450
#169COMPOSITIONS COMPRISING SPIRULINA COMPONENTS
#170A TUNABLE PHOSPHORYLATION-BASED FEEDBACK CONTROLLER OF MAMMALIAN GENE EXPRESSION
#171Application of RDR protein in tumor therapy
#172Ocular Compositions and Methods Thereof
#173COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#174Anti-inflammatory peptides and composition comprising the same
#175TREATMENT OF HYPERBILIRUBINEMIA
#176ENHANCED HYT-INDUCED PROTEIN DEGRADATION USING LIPID NANOPARTICLE DELIVERY
#177COMBINATION THERAPY OF MDNA55 AND A VASCULAR ENDOTHELIAL GROWTH FACTOR A (VEGF-A)
#178COMPOSITION FOR REGULATING OSTEOCLAST DIFFERENTIATION, AND USE THEREOF
#179USE OF FRUCTOSYLTRANSFERASE
#180COMPOSITION CONTAINING FUNCTIONAL BLACK SOYBEAN POWDER BIOCONVERTED BY USING BACILLUS ENZYMES AS ACTIVE INGREDIENT, AND USE THEREOF
#181Methods for Treating and Monitoring the Status of Cancer
#182COMPOSITION FOR PREVENTING OR TREATING NEUROMUSCULAR DISEASE, COMPRISING PRMT1 PROTEIN OR GENE ENCODING SAME
#183ENGINEERED PROBIOTICS FOR EXPRESSION OF FIBER-SYNTHESIZING ENZYMES IN GUT
#184METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#185METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#186TRANSPOSON, GENE TRANSFER SYSTEM AND METHOD OF USING THE SAME
#187Permanent Epigenetic Gene Silencing
#188PEPTIDES FOR TREATMENT AND PREVENTION OF NONALCOHOLIC FATTY LIVER DISEASE AND FIBROSIS
#189METHODS OF CYTOTOXIC GENE THERAPY TO TREAT TUMORS
#190METHODS AND COMPOSITIONS FOR TRANSDUCING HEMATOPOIETIC STEM AND PROGENITOR CELLS IN VIVO
#191AZAINDOLYLPYRIDONE AND DIAZAINDOLYLPYRIDONE COMPOUNDS
#192Methods of administering 3,4-diaminopridine
#193METHODS FOR INDUCING CELL DIVISION OF POSTMITOTIC CELLS
#194PREDICTING CANCER RELAPSE AND TREATMENT OF CANCER DISEASES
#195ALK POLYPEPTIDES AND METHODS OF USE THEREOF
#196Methods of administering 3,4-diaminopridine
#197GENE THERAPEUTICS FOR FIBRODYSPLASIA OSSIFICANS PROGRESSIVA
#198Anti-inflammatory peptides and composition comprising the same
#199BRK PEPTIDES AND METHODS OF USE
#200Treatment delivery system and method
#201DIAGNOSTIC METHODS FOR CANCER USING AXL DECOY RECEPTORS
#202ACTIVE DELIVERY OF NUCLEIC ACIDS AND PEPTIDES, METHODS AND USES
#203METHODS, DEVICES, AND SYSTEMS FOR TREATING LENS PROTEIN AGGREGATION DISEASES
#204Methods and Compositions to Target and Treat Macrophages
#205Compounds and Methods for Treating, Ameliorating, or Preventing Herpes Ocular Keratitis
#20628 KDA GST PROTEINS FROM SCHISTOSOMA FOR THE TREATMENT OF VASCULITIS
#207COMPOSITIONS AND METHODS FOR TREATING PULMONARY HYPERTENSION
#208ENZYME-MEDIATED DEPLETION OF ADENOSINE AND/OR METHYLTHIOADENOSINE
#209PEG LIPIDOID COMPOUNDS
#210MICRORNA-MEDIATED METHODS FOR REJUVENATING CNS GLIAL POPULATIONS
#211NEW USE OF CMTR1 HAVING SIRNA PRODUCTION AND FUNCTION ENHANCING ACTIVITY
#212METHODS FOR ANALYSIS OF SOMATIC MOBILE ELEMENTS, AND USES THEREOF
#213COMPOSITIONS AND METHODS FOR TREATING MYELIN DEFICIENCY BY REJUVENATING GLIAL PROGENITOR CELLS
#214BOTTOM-UP ASSEMBLY OF SYNTHETIC EXTRACELLULAR VESICLES
#215COMPOSITIONS AND METHODS FOR TREATMENT OF FAMILIAL HYPERCHOLESTEROLEMIA AND ELEVATED LOW-DENSITY LIPOPROTEIN CHOLESTEROL
#216COMBINATORIAL THERAPIES INCLUDING IMPLANTABLE DAMPING DEVICES AND BIOLOGIC THERAPEUTIC AGENTS FOR TREATING A CONDITION AND ASSOCIATED SYSTEMS AND METHODS OF USE
#217MICROBIAL CONSORTIA
#218USE OF CD83 IN COMBINATION THERAPIES
#219POLYMER WITH CATIONIC AND HYDROPHOBIC SIDE CHAINS
#220VIRAL VECTORS FOR TREATING NEUROGENIC DETRUSOR OVERACTIVITY
#221MICROENCAPSULATION OF NICOTINE FOR TOBACCOLESS ORAL ADMINISTRATION
#222N6-Methyladenosine Regulators in Uterine Fibroids
#223POLYNUCLEOTIDES ENCODING PORPHOBILINOGEN DEAMINASE FOR THE TREATMENT OF ACUTE INTERMITTENT PORPHYRIA
#224Nanoparticle Modification of Human Adipose-Derived Mesenchymal Stem Cells for Treating Brain Cancer and Other Neurological Diseases
#225ADVANCED MICROBIOME THERAPEUTICS ENGINEERED TO PRODUCE SEROTONIN IN VIVO
#226Methods of treating cancers having a BRCA1 and/or BRCA2 mutation(s)
#227RECOMBINANT THERAPEUTIC INTERVENTIONS FOR CANCER
#228Tricine and Citric Acid Lipids
#229METHODS AND COMPOSITIONS FOR DELIVERY OF AGENTS ACROSS THE BLOOD-BRAIN BARRIER
#230COMPOSITIONS AND METHODS FOR INDUCING IMMUNE TOLERANCE IN TRANSPLANTATION RECIPIENTS
#231COMPOSITIONS AND METHODS FOR COMPARTMENT-SPECIFIC CARGO DELIVERY
#232Methods and compositions for genomic integration
#233SUBCUTANEOUS DELIVERY OF MESSENGER RNA
#234ARYL AND HETEROARYL COMPOUNDS, AND THERAPEUTIC USES THEREOF IN CONDITIONS ASSOCIATED WITH THE ALTERATION OF THE ACTIVITY OF GALACTOCEREBROSIDASE
#235The Kinase NEK10 and Its Use in Treating and Diagnosing Bronchiectasis and Other Respiratory Disorders
#236Compositions targeting the interaction domain between p27KIP1 and Brk and methods of use thereof to inhibit p27 Y phosphorylation and cdk4 activity
#237USE OF PHOSPHORYLATED TAU AND P38GAMMA TO TREAT A NEUROLOGICAL CONDITION
#238Nucleobase Editors
#239Hydrodynamic Methods for Delivering Fluids to Kidney Tissues and Related Materials and Methods
#240Peptides and other agents for treating pain and increasing pain sensitivity
#241Methods and Compositions for Modulationg Heterochromatin Dysfunction, Genomic Instability, and Associate Conditions
#242Methods of Administering 3,4-Diaminopyridine
#243INHIBITING THE RNA METHYLTRANSFERASE METTL3 OR ITS INTERACTION WITH EIF3H TO SUPPRESS ONCOGENE TRANSLATION AND TUMORIGENESIS
#244Hydrogel composition, hydrogel biomedical material, method for facilitating regeneration of bone and manufacturing method of hydrogel composition
#245REGULATION OF RAN TRANSLATION BY PKR AND EIF2A-P PATHWAYS
#246NANOCOMPLEXES OF POLYANION-MODIFIED PROTEINS
#247Histone Deacytlase 6 Modulation of Titin Protein Mediated Cardiac Tissue Stiffness and Method for Same
#248Dry Powder Formulations for Messenger RNA
#249METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#250Methods for Treating Cancer That Has A Phosphatidylinositol 3,4,5-Trisphosphate Rac Exchange Factor 2 (PREX2) Protein Expressed Thereon
#251PEPTIDES AND COMPOSITIONS FOR TREATMENT OF JOINT DAMAGE
#252Novel RNA Composition and Production Method for Use in iPS Cell Generation
#253TGF-BETA SUPERFAMILY TYPE I AND TYPE II RECEPTOR HETEROMULTIMERS AND USES THEREOF
#254METHODS OF USING FLT3L-Fc FUSION PROTEINS
#255Compounds and methods for the targeted degradation of enhancer of zeste homolog 2 polypeptide
#256METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#257TREATMENT AND PREVENTION OF OCULAR NEURODEGENERATIVE DISORDER
#258METHODS FOR IMPROVED THERAPEUTIC USE OF RECOMBINANT AAV
#259ANC80 ENCODING SPHINGOLIPID-METABOLIZING PROTEINS FOR MITIGATING DISEASE-INDUCED TISSUE DAMAGE
#260COMPOSITIONS AND METHODS FOR DELIVERY OF RNA
#261REDUCING THE RISK OF MAJOR ADVERSE CARDIAC EVENTS
#262Anti-inflammatory peptides and composition comprising the same
#263APPLICATION OF TPK AS A TARGET IN ALZHEIMER'S DISEASE
#264METHODS OF CYTOTOXIC GENE THERAPY TO TREAT TUMORS
#265SYNTHETIC LIPID-LIKE MATERIALS FOR BRAIN DELIVERY
#266METHODS AND COMPOSITIONS INVOLVING TERT ACTIVATING THERAPIES
#267COMPOSITIONS DERIVED FROM HUMAN AMNION CELLS & RELATED METHODS
#268ASH1L inhibitors and methods of treatment therewith
#269Compositions Comprising Decarboxylated Cannabinoids
#270METHOD FOR THE MANUFACTURE OF A DOSAGE FORM WITH MUCOADHESIVE PROPERTIES FOR BUCCAL ADMINISTRATION OF BIOLOGICS
#271METHODS FOR TREATING RAN PROTEIN-ASSOCIATED NEUROLOGICAL DISEASES
#272NON-VIRAL MODIFICATION OF MESENCHYMAL STEM CELLS
#273DI-THIOESTER CATIONIC LIPIDS
#274NOVEL USE OF MPK38/MELK AS THERAPEUTIC AGENT FOR OBESITY OR METABOLIC DISEASES SPECIFIC TO MIDDLE-AGED MEN
#275FIBROBLAST CELL THERAPY FOR TREATMENT OF OSTEOPOROSIS
#276METHOD AND VEHICLE FOR DELIVERING AGENTS ACROSS THE BLOOD-BRAIN BARRIER
#277Pegylated capsule-degrading enzyme for the treatment of anthrax
#278CAMKK1 AS A NOVEL REGENERATIVE THERAPEUTIC
#279Pharmaceutical Compositions Comprising Integration-Promoting Peptides
#280THIOESTER CATIONIC LIPIDS
#281PRODUCTION AND USE OF EXTRACELLULAR VESICLE-CONTAINED ENAMPT
#282CHOLIX TOXIN-DERIVED FUSION MOLECULES FOR ORAL DELIVERY OF BIOLOGICALLY ACTIVE CARGO
#283METHODS FOR TREATING NEURODEGENERATIVE DISORDERS
#284MACROCYCLIC LIPIDS
#285NME INHIBITORS AND METHODS OF USING NME INHIBITORS
#286COMBINATION GMCI AND ATRI CANCER TREATMENT
#287COMPOSITIONS AND METHODS FOR DETOXIFYING BACTERIAL ENDOTOXINS
#288Method of treating aging-associated cognitive impairment by reducing CCR3
#289GMCI AND DDRI COMBINATION THERAPY FOR TREATING CANCER
#290COMPOSITIONS COMPRISING A TWEAK LIGAND AND METHODS OF USING SAME
#291ONCOLYTIC VIRUS WITH IMPROVED SAFETY AND ANTICANCER EFFECTS
#292Cleavable lipids
#293AUTOANTIBODIES AS BIOMARKER OF PARANEOPLASTIC ENCEPHALITIS ASSOCIATED WITH TESTICULAR CANCER
#294ABHD5 AND PARTIAL HDAC4 FRAGMENTS AND VARIANTS AS A THERAPEUTIC APPROACH FOR THE TREATMENT OF CARDIOVASCULAR DISEASES
#295B CELLS FOR IN VIVO DELIVERY OF THERAPEUTIC AGENTS AND DOSAGES THEREOF
#296METHODS OF TREATING IMBALANCE OF PLASMA LIPIDS LEVEL AND FATTY LIVER WITH M2C MACROPHAGES
#297Gene therapeutics for fibrodysplasia ossificans progressiva
#298CYSTINE CATIONIC LIPIDS
#299PIP4Ks SUPPRESS INSULIN SIGNALING AND ENHANCE IMMUNE FUNCTION THROUGH A CATALYTIC-INDEPENDENT MECHANISM
#300NUCLEIC ACID CONSTRUCT ENCODING Trk FRAGMENT AND USE THEREOF