21410 ⎘
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the administration regime
System comprising a nucleotide sequence encoding a volvox carteri light-activated ion channel protein (VCHR1)
#302Methods for increasing platelet count by inhibiting biliverdin IXβ reductase
#303BAG3 COMPOSITIONS AND METHODS
#304INTRANASAL THERAPEUTIC DELIVERY OF ADENO-ASSOCIATED VIRUS TO CENTRAL NERVOUS SYSTEM
#305Methods for modulating development and function of photoreceptor cells
#306REPEATED ADMINISTRATION OF LENTIVIRAL VECTORS TO RESPIRATORY CELLS
#307Thyroid stimulating hormone receptor peptides and uses thereof
#308PYRUVATE COMPOUNDS FOR TREATMENT OF PERIPHERAL NEUROPATHY
#309Toxicity management for anti-tumor activity of CARs
#310COMPOSITIONS AND METHODS FOR PROMOTING HOMOLOGY DIRECTED REPAIR
#311Polymer-iron oxide nano-complex, uses thereof and preparation method thereof
#312Toxicity management for anti-tumor activity of CARs
#313Method to achieve extended expression of DNA infused into liver
#314Immunoadsorption
#315ADMINISTRATION OF GROWTH FACTORS FOR THE TREATMENT OF CNS DISORDERS
#316Methods for creating a transgenic cell with microbubbles
#317TREATMENT WITH ANTI-EFNA4 ANTIBODY-DRUG CONJUGATES
#318ADENO-ASSOCIATED VIRUS FOR THERAPEUTIC DELIVERY TO CENTRAL NERVOUS SYSTEM
#319Systems, methods and compositions for optical stimulation of target cells
#320Therapeutic miRNAs for treating heart and skeletal muscle diseases
#321CENTRAL NERVOUS SYSTEM TARGETING POLYNUCLEOTIDES
#322Combination Therapy For Cancer
#323Efficient delivery of therapeutic molecules in vitro and in vivo
#324AAV-Based Gene Therapy
#325NANOVECTORS FOR PENETRATING BRAIN TUMOR TISSUES TO CONDUCT GENE THERAPY
#326Method for efficient delivery of therapeutic molecules in vitro and in vivo
#327System utilizing light-activated ion channel protein (VChR1) for optical stimulation of target cells
#328Engineered nucleic acids and methods of use thereof
#329Methods and materials for increasing viral vector infectivity
#330Systems and methods for nucleic acid expression in vivo
#331Vesicular stomatitis viruses
#332METHODS OF PERMITTING A SUBJECT TO RECEIVE MULTIPLE DOSES OF RECOMBINANT ADENO-ASSOCIATED VIRUS
#333Cancer Therapy
#334METHODS AND COMPOSITIONS FOR GENE DELIVERY TO ON BIPOLAR CELLS
#335Treatment of retinal degeneration using gene therapy
#336METHODS FOR ENHANCING THE DELIVERY OF ACTIVE AGENTS
#337Therapeutic miRNAs for treating heart and skeletal muscle diseases
#338Upconversion of light for use in optogenetic methods
#339System for electrically stimulating target neuronal cells of a living animal in vivo
#340OPTICAL TISSUE INTERFACE METHOD AND APPARATUS FOR STIMULATING CELLS
#341ENGINEERED NUCLEIC ACIDS AND METHODS OF USE THEREOF FOR NON-HUMAN VERTEBRATES
#342Treatment of neurological diseases using adeno-associated virus (AAV) comprising AAV-5 capsid proteins
#343MARKERS FOR LIPID METABOLISM
#344Method for optically controlling a neuron with a mammalian codon optimized nucleotide sequence that encodes a variant opsin polypeptide derived from natromonas pharaonis (NpHR)
#345Method for increasing expression of RNA-encoded proteins
#346Delivery of a therapeutic agent to the cerebral cortex by administering a viral vector by convection enhanced diffusion into the white matter of the brain
#347Pharmaceutical composition containing a stabilised mRNA optimised for translation in its coding regions
#348Pharmaceutical composition containing a stabilised mRNA optimised for translation in its coding regions
#349PHARMACEUTICAL COMPOSITION CONTAINING A STABILISED mRNA OPTIMISED FOR TRANSLATION IN ITS CODING REGIONS
#350Immunomodulating gene therapy
#351Foreign DNA surveillance protein
#352Methods for modulating development and function of photoreceptor cells
#353Administration of growth factors for the treatment of CNS disorders
#354System for optical stimulation of target cells
#355Elimination of immune responses to viral vectors
#356Matrix metalloproteinase cleavable protein polymers for cancer gene therapy
#357Pharmaceutical composition containing a stabilised mRNA optimised for translation in its coding regions
#358Pharmaceutical Composition and Method for the Treatment of Neurodegenerative Diseases, in Particular Amyotrophic Lateral Sclerosis
#359Methods and pharmaceutical compositions for the treatment of an ocular disease in a subject
#360Methods and compositions for increasing sialic acid production and treating sialic related disease conditions
#361Uniform field magnetization and targeting of therapeutic formulations
#362Upconversion of light for use in optogenetic methods
#363Mammalian codon optimized nucleotide sequence that encodes a variant opsin polypeptide derived from Natromonas pharaonis (NpHR)
#364Methods for therapy of neurodegenerative disease of the brain
#365Administration of growth factors for the treatment of CNS disorders
#366Methods for use of a specific anti-angiogenic adenoviral agent
#367Light-switchable gene expression system
#368Delivery of a gene therapy vector to the brain by convection-enhanced delivery
#369Method for vector delivery
#370Vesicular stomatitis viruses
#371Custom designed microbubble contrast agents and techniques of ultrasound delivery optimized for gene therapy
#372Uniform field magnetization and targeting of therapeutic formulations
#373Uniform field magnetization and targeting of therapeutic formulations
#374METHODS FOR THE TREATMENT OF TAY-SACHS DISEASE, SANDHOFF DISEASE, AND GM1-GANGLIOSIDOSIS
#375Optical based delivery of exogenous molecules to cells
#376METHODS AND COMPOSITIONS FOR INCREASING SIALIC ACID PRODUCTION AND TREATING SIALIC RELATED DISEASE CONDITIONS
#377Methods for intracellular delivery of nucleic acids
#378Uniform Field Magnetization and Targeting of Therapeutic Formulations
#379HIV vaccine formulations
#380Methods for transfecting nucleic acid into live cells
#381Cancer therapy
#382Methods for phototransfecting nucleic acids into live cells
#383Engineered nucleic acids and methods of use thereof
#384METHOD OF CONTROLLING INITIAL DRUG RELEASE OF siRNA FROM SUSTAINED-RELEASE IMPLANTS
#385Administration of growth factors for the treatment of CNS disorders
#386COMPOSITIONS AND METHODS FOR EX VIVO HEPATIC NUCLEIC ACID DELIVERY
#387Optogenetic method for generating an inhibitory current in a mammalian neuron
#388VIRAL VECTORS AND METHODS FOR PRODUCING AND USING THE SAME
#389METHOD FOR VECTOR DELIVERY
#390Regeneration of Pancreatic Islets and Reversal of Diabetes by Islet Transcription Factor Genes Delivered in Vivo
#391Delivery of DNA or RNA Via Gap Junctions from Host Cells to Target Cells and a Cell-Based Delivery System for Antisense or siRNA
#392PHARMACEUTICAL COMPOSITION CONTAINING A STABILISED mRNA OPTIMISED FOR TRANSLATION IN ITS CODING REGIONS
#393PARVOVIRAL CAPSID WITH INCORPORATED GLY-ALA REPEAT REGION
#394METHODS AND COMPOSITIONS FOR TARGETED DELIVERY OF GENE THERAPEUTIC VECTORS
#395Elimination of immune responses to viral vectors
#396Systems, methods and compositions for optical stimulation of target cells
#397PHARMACEUTICAL COMPOSITION CONTAINING A STABILISED MRNA OPTIMISED FOR TRANSLATION IN ITS CODING REGIONS
#398Delivery of DNA or RNA via gap junctions from host cells to target cells and a cell-based delivery system for antisense or siRNA
#399Immunomodulating gene therapy
#400Method for opening tight junctions
#401Use of microwave irradiation for delivery of macromolecules
#402Method and apparatus for device controlled gene expression for cardiac protection
#403Uniform field magnetization and targeting of therapeutic formulations
#404Widespread gene delivery to motor neurons using peripheral injection of AAV vectors
#405PHARMACEUTICAL COMPOSITION CONTAINING A STABILISED mRNA OPTIMISED FOR TRANSLATION IN ITS CODING REGIONS
#406VECTOR ENCODING THERAPEUTIC POLYPEPTIDE AND SAFETY ELEMENTS TO CLEAR TRANSDUCED CELLS
#407System for optical stimulation of target cells
#408Method for Using Lowstrength Electric Field Network (LSEN) and Immunosuppressive Strategies to Mediate Immune Responses
#409ACOUSTICALLY DELIVERING METHODS AND COMPOSITONS FOR REMOTE TREATMENT OF A TUMOR
#410REPEATED ADMINISTRATION OF LENTIVIRAL VECTORS TO RESPIRATORY CELLS
#411Growth hormone releasing hormone treatment to decrease cholesterol levels
#412Liver-directed gene therapy
#413COMPOSITION AND METHOD TO ALTER LEAN BODY MASS AND BONE PROPERTIES IN A SUBJECT
#414Use of nucleic acids with reduced pressure therapy
#415HIV VACCINE FORMULATIONS
#416Methods for treating pain
#417GENE THERAPY FOR NIEMANN-PICK DISEASE TYPE A
#418LIGHT ACTIVATED GENE TRANSDUCTION USING LONG WAVELENGTH ULTRAVIOLET LIGHT FOR CELL TARGETED GENE DELIVERY
#419SYSTEMS, METHODS AND COMPOSITIONS FOR OPTICAL STIMULATION OF TARGET CELLS
#420Enhanced retinal delivery of a nucleic acid through iontophoresis
#421Optical tissue interface method and apparatus for stimulating cells
#422Uniform field magnetization and targeting of therapeutic formulations
#423Method of achieving persistent Transgene expression
#424Methods and reagents for the enhancement of virus transduction in the bladder epithelium
#425Materials and methods for treating ocular-related disorders
#426REDUCING CULLING IN HERD ANIMALS GROWTH HORMONE RELEASING HORMONE (GHRH)
#427Methods of treating neoplasia with combination target cell-specific adenovirus, chemotherapy and radiation
#428Method and reagents for the enhancement of virus transduction in the bladder epithelium
#429METHOD OF MODULATING NEUTRALIZING ANTIBODIES FORMATION IN MAMMALS, AND USES THEREOF IN GENE THERAPY, ANIMAL TRANGENESIS AND IN FUNCTIONAL INACTIVATION OF ENDOGENOUS PROTEINS
#430Minimizing Metal Toxicity During Electroporation Enhanced Delivery of Polynucleotides
#431Gene introduction efficiency enhancer
#432Methods and reagents for the enhancement of virus transduction in the bladder epithelium
#433Methods and reagents for the enhancement of virus transduction in the bladder epithelium
#434Methods and reagents for the enhancement of virus transduction in the bladder epithelium
#435System for optical stimulation of target cells
#436Adenoviral Vector Compositions
#437Combinatorial Methods For Inducing Cancer Cell Death
#438Administration of growth factors for the treatment of CNS disorders
#439Cytokine-expressing cancer immunotherapy combinations
#440Delivery of DNA or RNA via gap junctions from host cells to target cells and a cell-based delivery system for antisense or siRNA
#441Therapeutic methods for nucleic acid delivery vehicles
#442Composition for transfection of DNA into the liver
#443Expression of zeta negative and zeta positive nucleic acids using a dystrophin gene
#444COMBINED TUMOR SUPPRESSOR GENE THERAPY AND CHEMOTHERAPY IN THE TREATMENT OF NEOPLASMS
#445Method and apparatus for modifying tissue to improve electrical stimulation efficacy
#446Glucocorticoid modulation of nucleic acid-mediated immune stimulation
#447Method and apparatus for device controlled gene expression for cardiac protection
#448Methods for therapy of neurodegenerative disease of the brain
#449Method of using a lead to regulate protein expression
#450Biologic device for regulation of gene expression and method therefor
#451Combined tumor suppressor gene therapy and chemotherapy in the treatment of neoplasms
#452Method of Enhancing Therapeutic Effect of Nucleic Acids
#453Method for gene transfer into the organelles of cells: direct gene transfer to mitochondria
#454Regulation of vascular endothelium using BMX tyrosine kinase
#455Wound healing method and kits
#456Methods for treating or preventing angiogenesis-dependent symptoms
#457Combination gene delivery vehicles
#458Direct DNA delivery to bone cells
#459Hiv vaccine formulations
#460Intravascular delivery of nucleic acid
#461Gene therapy with chimeric oligonucleotides delivered by a method comprising a step of iontophoresis
#462Methods of treating neoplasia with combinations of target cell-specific adenovirus and chemotherapy
#463Medical devices and methods for delivering compositions to cells
#464Methods for treating pain
#465Method of reducing side effects of cancer therapy using p53 recombinant adenovirus
#466Molecule-releasing apparatus and molecule-releasing medhod
#467Inhibition of gene expression by delivery of small interfering RNA to post-embryonic animal cells in vivo
#468Method and agent for treating vulnerable plaque
#469Compositions and methods for enhancing receptor-mediated cellular internalization
#470Process for delivering nucleic acids to cardiac tissue
#471Materials and methods for treating ocular-related disorders
#472Viral vectors and methods for producing and using the same
#473Therapeutic fusion protein transgenes
#474Coronary artery disease treatment
#475Intravascular delivery of nucleic acid
#476Intravascular delivery of non-viral nucleic acid
#477Combined tumor suppressor gene therapy and chemotherapy in the treatment of neoplasms
#478Methods for therapy of neurodegenerative disease of the brain
#479Gene delivery compositions and methods
#480Delivering genetic material to a stimulation site
#481Light activated gene transduction for cell targeted gene delivery in the spinal column
#482Controlled release polymer nanoparticle containing bound nucleic acid ligand for targeting
#483Pharmaceutical composition containing a stabilised mRNA optimised for translation in its coding regions
#484Treatments for ocular neovascularization
#485Immunization of large mammals with low doses of RNA
#486Nucleic acid-polypeptide compositions and methods of inducing exon skipping
#487Method for the treatment of malignancies
#488Method for the treatment of malignancies