21411 ⎘
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy Purification or manufacturing processes for gene therapy compositions
GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING GENETICALLY CORRECTED AUTOLOGOUS KERATINOCYTES
#2FORMULATIONS FOR AAV GENE THERAPY
#3MODIFIED LIGAND-GATED ION CHANNELS AND METHODS OF USE
#4CAPSID POLYPEPTIDES AND METHODS OF USE THEREOF
#5Lipid-Coated Nanoparticles
#6Benzaldehyde acetal acid-degradable amphiphilic lipid and self-assembling peptides
#7GENE THERAPY FOR TREATING PROPIONIC ACIDEMIA
#8COMPOSITIONS AND METHODS FOR TREATING CEP290-ASSOCIATED DISEASE
#9SUPER MINIMAL INVERTED TERMINAL REPEAT (ITR) SEQUENCES AND USES THEREOF
#10HYBRID PEPTIDE DENDRIMER SYSTEMS AND EXTRAHEPATIC DELIVERY
#11REVERSIBLE, COVALENT POLYNUCLEOTIDE CONDENSATION APPROACH FOR ENHANCED GENE DELIVERY
#12CHEMICALLY-MODIFIED ADENO-ASSOCIATED VIRUSES
#13GENE THERAPY
#14SILICA PARTICLES FOR ENCAPSULATING NUCLEIC ACIDS
#15A SYSTEM FOR AN OCULAR GENE THERAPY AND A PROCESS FOR PREPARING THEREOF
#16COMPOSITIONS AND METHODS FOR PROMOTING HOMOLOGY DIRECTED REPAIR
#17GENE EDITING OF CAR-T CELLS FOR THE TREATMENT OF T CELL MALIGNANCIES WITH CHIMERIC ANTIGEN RECEPTORS
#18GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING GENETICALLY CORRECTED AUTOLOGOUS KERATINOCYTES
#19COMPOSITIONS AND METHODS FOR TRANSIENT GENE THERAPY WITH ENHANCED STABILITY
#20Targeted CRISPR Delivery Platforms
#21NUCLEIC ACID COMPOSITIONS COMPRISING A MULTIVALENT ANION, SUCH AS AN INORGANIC POLYPHOSPHATE, AND METHODS FOR PREPARING, STORING AND USING THE SAME
#22TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE
#23Compositions and Methods for TTR Gene Editing and Treating ATTR Amyloidosis
#24Targeted CRISPR Delivery Platforms
#25DRY POWDER COMPOSITION COMPRISING LONG-CHAIN RNA
#26METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#27METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#28Lipid Nanoparticle Compositions and Methods for mRNA Delivery
#29METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS
#30NOVEL IMMUNOSTIMULATING VECTOR SYSTEM
#31THERAPEUTIC APPLICATIONS OF CPF1-BASED GENOME EDITING
#32DRY POWDER COMPOSITION COMPRISING LONG-CHAIN RNA
#33Lipid Nanoparticle Compositions and Methods for mRNA Delivery
#34DELIVERY AND USE OF THE CRISPR-CAS SYSTEMS, VECTORS AND COMPOSITIONS FOR HEPATIC TARGETING AND THERAPY
#35STABILIZED FORMULATIONS OF CHIMPANZEE ADENOVIRUS
#36METHODS AND COMPOSITIONS FOR THE TREATMENT OF RARE DISEASES
#37GENE EDITING OF CAR-T CELLS FOR THE TREATMENT OF T CELL MALIGNANCIES WITH CHIMERIC ANTIGEN RECEPTORS
#38GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING GENETICALLY CORRECTED AUTOLOGOUS KERATINOCYTES
#39CELL-TYPE SPECIFIC MEMBRANE FUSION PROTEINS
#40METHODS FOR FORMING POLYPLEXES
#41PROCESSES OF PREPARING MRNA-LOADED LIPID NANOPARTICLES
#42COMPOSITIONS AND SYSTEMS COMPRISING TRANSFECTION-COMPETENT VESICLES FREE OF ORGANIC-SOLVENTS AND DETERGENTS AND METHODS RELATED THERETO
#43COMPOSITIONS AND SYSTEMS COMPRISING TRANSFECTION-COMPETENT VESICLES FREE OF ORGANIC-SOLVENTS AND DETERGENTS AND METHODS RELATED THERETO
#44EXTRACELLULAR VESICLES FOR INHALATION
#45CAPSID VARIANTS AND METHODS OF USING THE SAME
#46SCALABLE PRODUCTION METHOD FOR AAV
#47CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS WITH BLUNTED INNATE IMMUNE RESPONSES
#48ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#49EVOLUTION OF TALENS
#50HSV AMPLICON PACKAGING SYSTEM USING ENGINEERED CELLS
#51PRODUCTION OF CIRCULAR POLYRIBONUCLEOTIDES IN A EUKARYOTIC SYSTEM
#52Methods and Compositions for Modifying a Mutant Dystrophin Gene in a Cell's Genome
#53METHODS OF PREPARATION OF NOVEL PAN TLR ANTAGONISTIC LIPOSOMAL-LNP FORMULATIONS AND USES THEREOF
#54COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS AND/OR VISION LOSS
#55CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS WITH BLUNTED INNATE IMMUNE RESPONSES
#56Method of Increasing the Function of an AAV Vector
#57RAPID DESIGN, BUILD, TEST, AND LEARN TECHNOLOGIES FOR IDENTIFYING AND USING NON-VIRAL CARRIERS
#58METHODS FOR PREPARATION OF PLASMID DNA/LIPID PARTICLES WITH DEFINED SIZE FOR IN VITRO AND IN VIVO TRANSFECTION
#59Gene therapy for recessive dystrophic epidermolysis bullosa using genetically corrected autologous keratinocytes
#60AMINO ALCOHOL IONIZABLE LIPIDS
#61AMINO ALCOHOL IONIZABLE LIPIDS
#62METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#63FORMULATIONS FOR SUPRACHOROIDAL ADMINISTRATION SUCH AS GEL FORMULATIONS
#64PERFUSION-GUIDED GENE THERAPY FOR IMPROVING CANCER TREATMENT
#65METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#66ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#67Lipid nanoparticle compositions and methods for mRNA delivery
#68ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#69LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#70METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#71Lipid nanoparticle compositions and methods for MRNA delivery
#72Lipid nanoparticle compositions and methods for MRNA delivery
#73METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#74Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#75COMPOSITION AND METHODS OF GENOME EDITING OF B-CELLS
#76EXOSOMES COMPRISING THERAPEUTIC POLYPEPTIDES
#77Treating metastatic cancer and model systems for metastatic disease
#78METHODS FOR THE TREATMENT OF INFLAMMATORY JOINT DISEASE
#79METHOD FOR SPECIFICALLY EDITING GENOMIC DNA AND APPLICATION THEREOF
#80COMPOSITIONS AND METHODS FOR TREATING MACULAR DYSTROPHY
#81Methods and Compositions for Treatment of Disorders and Diseases Involving RDH12
#82Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#83SCALABLE PRODUCTION METHOD FOR AAV
#84Compositions and systems comprising transfection-competent vesicles free of organic-solvents and detergents and methods related thereto
#85NUCLEIC ACID LOADED RED BLOOD CELL EXTRACELLULAR VESICLES
#86PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF
#87Methods and Compositions for Treatment of Disorders and Diseases Involving RDH12
#88Methods and Compositions for Treatment of Disorders and Diseases Involving RDH12
#89PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF
#90COMPOSITIONALLY DEFINED PLASMID DNA/POLYCATION NANOPARTICLES AND METHODS FOR MAKING THE SAME
#91Targeted CRISPR Delivery Platforms
#92Dry powder composition comprising long-chain RNA
#93Method for delivering RNA to neurons to treat herpes infections
#94Lipid nanoparticle compositions and methods for mRNA delivery
#95ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#96LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#97NANOPARTICLE COMPLEX FOR TREATING DISEASES AND METHOD FOR MANUFACTURING THE SAME
#98Rapid design, build, test, and learn technologies for identifying and using non-viral carriers
#99Adeno-associated virus virions with variant capsid and methods of use thereof
#100Adeno-associated virus virions with variant capsid and methods of use thereof
#101METHODS FOR THE TREATMENT OF INFLAMMATORY JOINT DISEASE
#102Use of Thermostable RNA Polymerases to Produce RNAs Having Reduced Immunogenicity
#103COMPOSITIONS AND METHODS FOR TREATING CEP290-ASSOCIATED DISEASE
#104Allele-specific inactivation of mutant HTT via gene editing at coding region single nucleotide polymorphisms
#105RECOMBINANT AD35 VECTORS AND RELATED GENE THERAPY IMPROVEMENTS
#106ENGINEERED NUCLEASES USEFUL FOR TREATMENT OF HEMOPHILIA A
#107RAAV WITH CHEMICALLY MODIFIED CAPSID
#108GENE THERAPY USING GENETICALLY MODIFIED VIRAL VECTORS
#109Dry powder composition comprising long-chain RNA
#110CONSTRUCTS AND METHODS FOR DELIVERING MOLECULES VIA VIRAL VECTORS WITH BLUNTED INNATE IMMUNE RESPONSES
#111Compositions and systems comprising transfection-competent vesicles free of organic-solvents and detergents and methods related thereto
#112Methods and Compositions for Treatment of Disorders and Diseases Involving RDH12
#113Methods and Compositions for Treatment of Disorders and Diseases Involving RDH12
#114Nanoparticles comprising protein-polynucleotide complexes and for delivering protein based complexes
#115Lipid nanoparticle compositions and methods for mRNA delivery
#116LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#117Lipid nanoparticle compositions and methods for MRNA delivery
#118CELL PROCESSING UNIT, CELL PROCESSING SYSTEM AND METHODS OF USE THEREOF
#119Lipid nanoparticle compositions and methods for mRNA delivery
#120METHODS FOR FORMING POLYPLEXES
#121METHODS TO TREAT MITOCHONDRIAL-ASSOCIATED DYSFUNCTIONS OR DISEASES
#122Compositions and methods for promoting homology directed repair
#123CELL PROCESSING DEVICE CELL PROCESSING SYSTEM AND METHODS OF USE THEREOF
#124Drug Delivery Particle and Method for Producing the Same
#125Lipid nanoparticle compositions and methods for mRNA delivery
#126COMBINATION THERAPY FOR TREATING MUSCULAR DYSTROPHY
#127Evolution of TALENs
#128INHALATION POWDER MEDICINE, EVALUATION METHOD THEREOF, AND USE THEREOF
#129NUCLEIC ACID MOLECULES CONTAINING SPACERS AND METHODS OF USE THEREOF
#130Exosomes Comprising RNA Therapeutics
#131RECOMBINANT ADENO-ASSOCIATED VIRUS PARTICLE PURIFICATION COMPRISING AN AFFINITY PURIFICATION STEP
#132Smart multidosing
#133Vector for gene silencing and replacement and methods of use thereof
#134Extracellular vesicles for inhalation
#135Lipid nanoparticle compositions and methods for mRNA delivery
#136Compositions and methods for transient gene therapy with enhanced stability
#137GENE THERAPY FOR TREATING FAMILIAL HYPERCHOLESTEROLEMIA
#138Adeno-associated virus virions with variant capsid and methods of use thereof
#139GENE THERAPY FOR TREATING PROPIONIC ACIDEMIA
#140rAAV with chemically modified capsid
#141Processes of preparing mRNA-loaded lipid nanoparticles
#142CAPSID-MODIFIED, RAAV3 VECTOR COMPOSITIONS AND METHODS OF USE IN GENE THERAPY OF HUMAN LIVER CANCER
#143COMBINATORIAL GENE THERAPY
#144Immunostimulating vector system
#145Nucleic acid loaded extracellular vesicles
#146Modified ligand-gated ion channels and methods of use
#147RAAV with chemically modified capsid
#148Use of Syncytin for Targeting Drug and Gene Delivery to Lung Tissue
#149Use of thermostable RNA polymerases to produce RNAs having reduced immunogenicity
#150Lipid nanoparticle compositions and methods for mRNA delivery
#151Dry Transfection Compositions and Methods for Making and Using the Same
#152METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#153CAPSID-MODIFIED RAAV VECTORS AND METHODS OF USE
#154Dry powder composition comprising long-chain RNA
#155Scalable manufacturing platform for viral vector purification and viral vectors so purified for use in gene therapy
#156Delivery and use of the CRISPR-CAS systems, vectors and compositions for hepatic targeting and therapy
#157Scalable production method for AAV
#158Dry powder composition comprising long-chain RNA
#159Adenoviral Polypeptide IX Increases Adenoviral Gene Therapy Vector Productivity and Infectivity
#160Lipid nanoparticle compositions and methods for mRNA delivery
#161Method
#162Method of increasing the function of an AAV vector
#163Evolution of TALENs
#164Analytical HPLC methods
#165ISOLATION OF EXTRACELLULAR VESICLES (EVS) FROM RED BLOOD CELLS FOR GENE THERAPY
#166DELIVERY OF A GENE-EDITING SYSTEM WITH A SINGLE RETROVIRAL PARTICLE AND METHODS OF GENERATION AND USE
#167METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#168EXTRACELLULAR VESICLES FOR AGENT DELIVERY
#169NUCLEIC ACID-CATIONIC POLYMER COMPOSITIONS AND METHODS OF MAKING AND USING THE SAME
#170METHODS FOR THE TREATMENT OF INFLAMMATORY JOINT DISEASE
#171LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#172Nucleic acid application primers
#173NOVEL METHOD FOR GENE THERAPY USING INTRANASAL ADMINISTRATION OF GENETICALLY MODIFIED VIRAL VECTORS
#174Dry powder composition comprising long-chain RNA
#175Factor IX encoding nucleotides
#176Factor IX encoding nucleotides
#177Electroporation, developmentally-activated cells, pluripotent-like cells, cell reprogramming and regenerative medicine
#178Lyophilized pharmaceutical compositions for naked DNA gene therapy
#179METHODS FOR DETERMINING POTENCY OF ADENO-ASSOCIATED VIRUS PREPARATIONS
#180Method for the treatment of malignancies
#181GENE EDITING OF CAR-T CELLS FOR THE TREATMENT OF T CELL MALIGNANCIES WITH CHIMERIC ANTIGEN RECEPTORS
#182RAAV with chemically modified capsid
#183Recombinant adeno-associated virus particle purification comprising an affinity purification step
#184Gene therapy for recessive dystrophic epidermolysis bullosa using genetically corrected autologous keratinocytes
#185Formulation
#186Targeted CRISPR Delivery Platforms
#187CRISPRs IN SERIES TREATMENT
#188NATURAL KILLER T (NKT) CELLS COMPRISING ENGINEERED T CELL RECEPTORS
#189Lipid nanoparticle compositions and methods for mRNA delivery
#190SCALABLE MANUFACTURING PLATFORM FOR VIRAL VECTOR PURIFICATION AND VIRAL VECTORS SO PURIFIED FOR USE IN GENE THERAPY
#191Method of Encapsulating a Nucleic Acid in a Lipid Nanoparticle Host
#192Adenoviral Polypeptide IX Increases Adenoviral Gene Therapy Vector Productivity and Infectivity
#193COMPOSITIONS AND METHODS FOR TREATING MACULAR DYSTROPHY
#194Endosomolytic agents for gene therapy
#195Compositions and methods for mitochondrial genome editing
#196B-CELL-MIMETIC CELLS
#197Seeding An Adherent Cell Bioreactor With Non-Adherent Cells Increases Seeding Density Limit And Reduces Required Expansion Time
#198Nanoparticles comprising protein-polynucleotide complexes and for delivering protein based complexes
#199COMPOSITION AND METHODS OF GENOME EDITING OF B-CELLS
#200Process for recovering viral products using functionalised chromatography media
#201Method for delivering RNA to neurons to treat herpes infections
#202Vector for gene silencing and replacement and methods of use thereof
#203Method of increasing the function of an AAV vector
#204Adeno-associated virus particle with mutated capsid and methods of use thereof
#205Compositions and methods for treating CEP290-associated disease
#206GENE EDITING AND TARGETED TRANSCRIPTIONAL MODULATION FOR ENGINEERING ERYTHROID CELLS
#207Lipid nanoparticle compositions and methods for mRNA delivery
#208BCL11A HOMING ENDONUCLEASE VARIANTS, COMPOSITIONS, AND METHODS OF USE
#209Gene therapy
#210Dependent Component Genome Editing Gene Drives
#211Lipid nanoparticle compositions and methods for mRNA delivery
#212Modified ligand-gated ion channels and methods of use
#213Treating metastatic cancer and model systems for metastatic disease
#214METHODS AND COMPOSITIONS FOR THE TREATMENT OF RARE DISEASES
#215Treatment And/Or Prevention Of DNA-Triplet Repeat Diseases Or Disorders
#216Compositions and methods of replication deficient adenoviral vectors for vaccine applications
#217Exosomes comprising therapeutic polypeptides
#218GENE THERAPY FOR THE TREATMENT OF ALDEHYDE DEHYDROGENASE DEFICIENCY
#219Means and methods to treat dystonia
#220Method of engineering drug-specific hypersensitive t-cells for immunotherapy by gene inactivation
#221Therapeutic applications of CPF1-based genome editing
#222Methods and compositions for treatment of disorders and diseases involving RDH12
#223NANOPARTICLES COMPRISING PROTEIN-POLYNUCLEOTIDE COMPLEXES AND FOR DELIVERING PROTEIN BASED COMPLEXES
#224Engineered nucleases useful for treatment of hemophilia A
#225GENERATION OF GENETICALLY ENGINEERED ANIMALS BY CRISPR/CAS9 GENOME EDITING IN SPERMATOGONIAL STEM CELLS
#226Dry powder composition comprising long-chain RNA
#227TREATMENT OF NEUROPATHY WITH DNA CONSTRUCT EXPRESSING HGF ISOFORMS WITH REDUCED INTERFERENCE FROM GABAPENTINOIDS
#228Nanocapsule delivery system for ribonucleoproteins
#229METHODS AND COMPOSITIONS UTILIZING CPF1 FOR RNA-GUIDED GENE EDITING
#230SCALABLE PRODUCTION METHOD FOR AAV
#231Isolation of extracellular vesicles (EVs) from red blood cells for gene therapy
#232Immunostimulating vector system
#233Methods and compositions for modifying a mutant dystrophin gene in a cell's genome
#234MATERIALS AND METHODS FOR TREATMENT OF SEVERE COMBINED IMMUNODEFICIENCY (SCID) OR OMENN SYNDROME
#235Gene therapy for treating familial hypercholesterolemia
#236Engineered Cells Expressing Multiple Immunomodulators and Uses Thereof
#237Use of common gamma chain cytokines for the visualization, isolation and genetic modification of memory T lymphocytes
#238Method for determining presence or absence of suffering from malignant lymphoma or leukemia, and agent for treatment and/or prevention of leukemia
#239Method for the treatment of malignancies
#240Personalized medicine therapeutic MiniCircle
#241Recombinant Influenza Viruses for Vaccines and Gene Therapy
#242COMPOSITIONS AND METHODS FOR PROMOTING HOMOLOGY DIRECTED REPAIR
#243Evolution of TALENs
#244Capsid-modified, RAAV3 vector compositions and uses in gene therapy of human liver cancer
#245Compositions related to rna in circularized form
#246NUCLEIC ACID-CATIONIC POLYMER COMPOSITIONS AND METHODS OF MAKING AND USING THE SAME
#247Intervention for tendinopathy
#248Dry powder composition comprising long-chain RNA
#249Smart car devices, DE car polypeptides, side CARs and uses thereof
#250Nucleic acid molecules containing spacers outside ITR
#251Method of increasing the function of an AAV vector
#252EXCIPIENTS FOR USE IN ADENO-ASSOCIATED VIRUS PHARMACEUTICAL FORMULATIONS AND PHARMACEUTICAL FORMULATIONS MADE THEREWITH
#253Method for purifying viral vectors
#254Capsid modified rAAV vectors and methods of use
#255Extracellular vesicles for agent delivery
#256Poly(Beta-Amino Ester)s With Additives for Drug Delivery
#257Scalable manufacturing process to produce recombinant lentiviral vectors in serum-free suspension cell culture system
#258Method for producing therapeutic corneal endothelial substitute cell sphere
#259METHODS OF IDENTIFYING ANTIGENS FOR VACCINES
#260Lipid nanoparticle compositions and methods for MRNA delivery
#261CONDITIONAL CYTOTOXIC GENE THERAPY VECTOR FOR SELECTABLE STEM CELL MODIFICATION FOR ANTI HIV GENE THERAPY
#262Messenger RNA nanoparticles and preparation method therefor
#263Method of encapsulating a nucleic acid in a lipid nanoparticle host
#264Virus Purification
#265Treatment of lysosomal storage diseases
#266Drug delivery particle and method for producing the same
#267Engineered cells expressing multiple immunomodulators and uses thereof
#268Virus purification
#269Seeding An Adherent Cell Bioreactor With Non-Adherent Cells Increases Seeding Density Limit And Reduces Required Expansion Time
#270In vivo Gene Engineering with Adenoviral Vectors
#271Lyophilized lentiviral vector particles, compositions and methods
#272Gene therapy to prevent reactions to allergens
#273Methods for genetic modification of stem cells
#274DRY TRANSFECTION COMPOSITIONS AND METHODS FOR MAKING AND USING THE SAME
#275Methods for the treatment of inflammatory joint disease
#276Constructs and methods for delivering molecules via viral vectors with blunted innate immune responses
#277Scalable manufacturing platform for viral vector purification and viral vectors so purified for use in gene therapy
#278Nucleic acid-encapsulating polymer micelle complex and method for producing same
#279Nanocomplex containing amphipathic peptide useful for efficient transfection of biomolecules
#280Delivery and use of the CRISPR-Cas systems, vectors and compositions for hepatic targeting and therapy
#281DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR TARGETING AND MODELING DISEASES AND DISORDERS OF POST MITOTIC CELLS
#282Recombinant influenza viruses for vaccines and gene therapy
#283Capsid-modified rAAV vectors and methods of use
#284Drug delivery system and method
#285Scalable production method for AAV
#286Vectors comprising stuffer/filler polynucleotide sequences and methods of use
#287Compositions and Methods for Parkinson's Disease Treatment by BDNF-flag Gene Transfer through Neurotensin Polyplex to Nigral Dopamine Neuro
#288Automated generation of genetically modified stem cells
#289Use of common γ chain cytokines for the visualization, isolation and genetic modification of memory T lymphocytes
#290Reduction stimulus-responsive gene delivery system and preparation and application thereof
#291EXCIPIENTS FOR USE IN ADENO-ASSOCIATED VIRUS PHARMACEUTICAL FORMULATIONS, AND PHARMACEUTICAL FORMULATIONS MADE THEREWITH
#292Recombinant influenza vectors with tandem transcription units
#293Method of increasing the function of an AAV vector
#294Avian adenoassociated virus and uses thereof
#295Long lasting drug formulations
#296SCALABLE MANUFACTURING PROCESS TO PRODUCE RECOMBINANT LENTIVIRAL VECTORS IN SERUM-FREE SUSPENSION CELL CULTURE SYSTEM
#297Process for preparing purified nucleic acid and the use thereof
#298Bovine adeno-associated viral (BAAV) vector and uses thereof
#299Reassortant influenza viruses for vaccines
#300COMPOSITIONS AND METHODS FOR DELIVERING NUCLEIC ACID TO A CELL