109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
ADAM32 GENE IN THE DIAGNOSIS AND TREATMENT OF LUNG ADENOCARCINOMA
#302COMPOSITIONS AND METHODS FOR TREATING PANCREATIC CANCER
#303MODIFIED SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF
#304MODULAR RNA DELIVERY PLATFORMS AND METHODS OF THEIR USE
#305SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#306COMPOUNDS AND METHODS FOR REDUCING PRION EXPRESSION
#307COMPOSITIONS AND METHOD FOR THE TREATMENT OF X-LINKED DYSTONIA PARKINSONISM
#308Antisense Nucleic Acids for Use in the Treatment for LMNA Mutation Carriers
#309METHODS AND COMPOSITIONS FOR SELECTIVELY ELIMINATING CELLS OF INTEREST
#310COMPOSITIONS AND METHODS FOR THE TREATMENT OF CANCER USING A CD8 ENGINEERED T CELL THERAPY
#311METHODS AND COMPOSITIONS FOR WOUND HEALING
#312ANTIBODY-DRUG CONJUGATE WITH IMPROVED THERAPEUTIC WINDOW
#313APPLICATION OF COMPOUND OR TRADITIONAL CHINESE MEDICINE EXTRACT IN PREPARATION OF NUCLEIC ACID DELIVERY AGENT, AND RELATED PRODUCTS
#314ROTAVIRUS VACCINES
#315SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#316IONIZABLE LIPID CONTAINING BIODEGRADABLE DISULFIDE BOND AND LIPID NANOPARTICLES COMPRISING SAME
#317OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#318METHODS OF DIAGNOSING AND TREATING ALZHEIMER'S DISEASE
#319WNT-MODULATING GENE SILENCERS AS BONE ANABOLIC THERAPY FOR OSTEOPOROSIS AND CRITICAL-SIZED BONE DEFECT
#320DNA ASSEMBLY
#321Splint nucleic acid molecule for cyclizing single-stranded nucleic acid molecule and use thereof
#322Methods and Compositions for Adar-Mediated Editing
#323ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES
#324ADVANCED RNA TARGETING (ARNATAR)
#325Compositions and Methods for Inhibition of Factor XII Gene Expression
#326RNA INTERFERENCE OLIGONUCLEOTIDES FOR INHIBITING PERINEURONAL NETWORK FORMATION
#327SMALL ACTIVATING RNA (saRNA) CAPABLE OF ACTIVATING CCAAT ENHANCER BINDING PROTEIN ALPHA (CEBPA) GENE, AND DELIVERY SYSTEM AND USE THEREOF
#328NUCLEIC ACID COMPOUNDS
#329COMPOSITION AND METHODS FOR TRANSGENE INSERTION
#330SYSTEMS FOR CELL PROGRAMMING AND METHODS THEREOF
#331Compositions and methods for improved malonyl-CoA biosynthesis using 2-stage dynamic metabolic control
#332ENHANCED TRIACYLGLYCEROL PRODUCTIVITY AND EXTRACTABILITY IN AN ENGINEERED MICROALGA
#333EPO RECEPTOR AGONISTS AND ANTAGONISTS
#334RNA-DNA FUSOMERS AND METHODS OF USE THEREOF
#335DOUBLE-STRANDED RNA COMPRISING NUCLEOTIDE ANALOG CAPABLE OF REDUCING OFF-TARGET TOXICITY
#336METHODS OF IMPROVING SYSTEMIC DISEASE OUTCOMES BY INHIBITION OF ZHX2
#337CELL-PENETRATING PEPTIDES
#338IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#339METHODS FOR MANUFACTURING AND USING EXTRACELLULAR VESICLES
#340MICROSTRUCTURE FOR PREVENTION AND TREATMENT OF OBESITY AND OBESITY-DERIVED TYPE 2 DIABETES, COMPRISING COMPLEX OF GENE AND ADIPOCYTE-TARGETING GENE CARRIER
#341DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTIC APPLICATIONS
#342GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#343PROTAC-CID SYSTEMS FOR USE IN MULTIPLEX GENE REGULATION
#344LOX3 GENE MODULATION AND ARMYWORM TOLERANCE
#345DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS FOR RNA INTERFERENCE AND METHODS RELATING THERETO
#346SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#347NOVEL RNA THERAPEUTICS AND USES THEREOF
#348HMGB1 EXPRESSION REGULATOR, PROPHYLACTIC AGENT OR THERAPEUTIC AGENT FOR ACUTE LUNG INJURY, ACUTE RESPIRATORY DISTRESS SYNDROME, OR SEPSIS, OR METHOD OF AMELIORATING SAME
#349METHODS OF USING EXTRACELLULAR VESICLE-ASO TARGETING STAT6
#350COMPOSITIONS AND METHODS FOR TREATING DISEASES ASSOCIATED WITH PATHOGENIC FUS VARIANTS
#351Gene constructs for silencing alpha-synuclein and uses thereof
#352GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#353MUSCLE-TARGETING COMPLEXES AND USES THEREOF
#354MONOMERS AND METHODS FOR SYNTHESIS OF MODIFIED OLIGONUCLEOTIDES
#355GENE THERAPY FOR AADC DEFICIENCY
#356DELIVERY, USE AND THERAPEUTIC APPLICATIONS OF THE CRISPR-CAS SYSTEMS AND COMPOSITIONS FOR HBV AND VIRAL DISEASES AND DISORDERS
#357NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON SKIPPING
#358PRNP RNAi AGENTS
#359COMPOSITIONS AND METHODS FOR PROMOTING LIVER REGENERATION BY GENE EDITING IN METABOLIC LIVER DISEASE
#360THREOSE NUCLEIC ACID ANTISENSE OLIGONUCLEOTIDES AND METHODS THEREOF
#361Selective Antisense Compounds and Uses Thereof
#362COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
#363MIR449A AS A THERAPEUTIC FOR NEURODEGENERATIVE DISORDERS
#364NUCLEIC ACID COMPOUNDS
#365METHODS AND COMPOSITIONS FOR INHIBITION OF IRF4
#366THERAPEUTIC AGENT FOR CANCER, TESTING ASSISTANCE METHOD, AND SCREENING METHOD FOR THERAPEUTIC AGENT
#367EDITABLE CELL LINES
#368METHODS AND PRODUCTS FOR GENETIC ENGINEERING
#369COMBINATION OF ENGINEERED NATURAL KILLER (NK) CELLS AND ANTIBODY THERAPY AND RELATED METHODS
#370PRODUCTION OF IMMUNE CELLS
#371METHODS FOR AFFECTING TISSUE-RESIDENT T CELLS
#372RIBOZYMES
#373METHOD OF GENETICALLY RECOMBINING LACTIC ACID BACTERIA AND GRAM-POSITIVE BACTERIA USING CRISPR/CAS SYSTEM
#374Linkage Modified Oligomeric Compounds and Uses Thereof
#375COMPOSITIONS AND METHODS FOR CONTROL OF PSEUDOGYMNOASCUS DESTRUCTANS
#376Oligomeric Compounds Comprising Bicyclic Nucleotides and Uses Thereof
#377NUCLEIC ACID COMPOUNDS
#378OLIGONUCLEOTIDES
#379TREATMENT OF MS4A4E RELATED DISEASES AND DISORDERS
#380NON-CODING RNA SEQUENCES CAPABLE OF INCREASING THE EXPRESSION OF CHD8 AND CHD2 PROTEINS
#381Compositions and Methods for Treating FUS Associated Diseases
#382COMPOSITION COMPRISING TAF10 INHIBITOR FOR PREVENTING OR TREATING COLORECTAL CANCER
#383CYCLIC PHOSPHONATE-MODIFIED NUCLEOTIDE
#384COMPOSITIONS AND METHODS INVOLVING ADGRG6
#385CHIMERIC PEPTIDES FOR ANTISENSE DELIVERY
#386COMPOSITIONS AND METHODS FOR NON-GENOTOXIC CONDITIONING
#387POLYMER NANOPARTICLE COMPOSITIONS FOR NON-VIRAL GENE DELIVERY
#388SCREENING METHODS FOR RNA-CONTROLLING COMPOUNDS
#389GENE EDITING SYSTEM FOR TREATING DUCHENNE MUSCULAR DYSTROPHY, AND METHOD OF TREATING DISEASE USING SAME
#390METHODS AND COMPOSITIONS FOR PRODUCING SELF-AMPLIFYING RNA FOR GENE SILENCING IN PLANTS
#391RNA VECTORS WITH HAIRPIN-LIKE INSERTS
#392COMPOSITIONS AND METHODS FOR INDUCED TISSUE REGENERATION IN MAMMALIAN SPECIES
#393MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#394POLYNUCLEIC ACID MOLECULES TARGETING AGT AND USES THEREOF
#395ANTISENSE OLIGONUCLEOTIDES FOR TARGETING PROGRANULIN
#396MODIFIED U7 SNRNA CONSTRUCT
#397COMPOSITIONS FOR AND METHODS OF GENE EDITING
#398Promoters And Compositions
#399TARGETED REPLACEMENT OF ENDOGENOUS T CELL RECEPTORS
#400MINIGENE THERAPY
#401MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#402MRNA COMPOSITION FOR REGULATING MRNA TRANSLATION COMPRISING MRNA AND ANTISENSE OLIGONUCLEOTIDE COMPLEMENTARY TO PORTION OF THE MRNA
#403SHIELDED SMALL NUCLEOTIDES FOR INTRACELLULAR BARCODING
#404NANOPARTICLE COMPOSITIONS CONTAINING SUGAR FUNCTIONALIZED NUCLEIC ACID CARRIERS
#405RNA-GUIDED GENOME RECOMBINEERING AT KILOBASE SCALE
#406L-RNA APTAMER-ANTISENSE OLIGONUCLEOTIDE CONJUGATES AND USES THEREOF
#407DUAL-ACTING siRNA BASED MODULATION OF C9orf72
#408Antisense Compounds Targeted to CLN3 and Uses Thereof
#409MODIFIED ANTISENSE OLIGONUCLEOTIDES TARGETING FOXG1
#410MODIFIED U7 SNRNA CONSTRUCT
#411TARGETING MUC1-C WITH A NOVEL ANTISENSE OLIGONUCLEOTIDE FOR THE TREATMENT OF CANCER
#412COMPOSITION FOR TREATING CANCER
#413FUNCTIONAL NUCLEIC ACID MOLECULE
#414TARGETING ARHGAP5 GENE FUNCTION IN CANCER WITH ARHGAP35 ALTERATION
#415Modified Compounds and Uses Thereof
#416Ligand-Modified Oligonucleotides
#417DELIVERING GENES TO THE BRAIN ENDOTHELIUM TO TREAT LYSOSOMAL STORAGE DISORDER-DERIVED NEUROPATHOLOGY
#418COMPOSITIONS COMPRISING PLN-TARGETING ANTI-TRANSFERRIN RECEPTOR ANTIBODY-POLYNUCLEOTIDES AND METHODS OF USE THEREOF TO TREAT CARDIOMYOPATHY
#419VIRAL VECTOR PRODUCTION
#420CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#421Linkage Modified Oligomeric Compounds and Uses Thereof
#422COMPOSITIONS AND METHODS FOR TREATMENT OF MICROSATELLITE DNA EXPANSION DISORDERS
#423TARGETING MICRO RNA FOR TREATMENT OF HEART FAILURE WITH PRESERVED EJECTION FRACTION (HFPEF)
#424GENETIC SEQUENCE-CARBOHYDRATE CONJUGATES FOR ENHANCED LIVER- AND KIDNEY-SPECIFIC TARGETING
#425Antisense Oligonucleotide for Targeting Progranulin
#426SYNTHETIC INTRONS FOR TARGETED GENE EXPRESSION
#427ARTIFICIAL NUCLEIC ACID FOR INDUCING SPECIFIC THREE-DIMENSIONAL STRUCTURE
#428MODIFIED NUCLEIC ACID CONJUGATES
#429LEUKEMIA TREATMENT
#430CRISPR/Cas9-Mediated Exon-Skipping Approach for USH2A-Associated Usher Syndrome
#431EXTRACELLULAR VESICLES COMPRISING SMALL INTERFERING RNA
#432WIDE RANGE SYNTHETIC PEPTIDE NUCLEIC ACIDS AND THEIR APPLICATIONS
#433METHOD FOR REPAIRING HAIR CYCLE-RELATED GENES AND METHOD FOR TREATING HAIR CYCLE-RELATED DISEASES USING MIR-520D-5P
#434COMPOSITION AND METHOD FOR TREATMENT OF LCA10 USING RNA-GUIDED NUCLEASE
#435CELLS ENGINEERED WITH AN HLA-E AND HLA-G TRANSGENE
#436TREATMENT OF AUTOIMMUNE DISEASES WITH ENGINEERED IMMUNE CELLS
#437THROMBOMODULIN PROTEIN AND MIRNA FOR PREVENTING OR TREATING OSTEOATHRITIS
#438COMPOSITIONS AND METHODS FOR THE MODULATION OF MITOPHAGY FOR USE IN TREATMENT OF MITOCHONDRIAL DISEASE
#439APPLICATION OF COMPOUND OR TRADITIONAL CHINESE MEDICINE EXTRACT IN PREPARATION OF NUCLEIC ACID DELIVERY AGENT AND RELATED PRODUCTS THEREOF
#440COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#441COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#442COMPOSITIONS AND METHODS FOR NUCLEIC ACID TRANSFER
#443METHOD AND MEANS TO DELIVER miRNA TO TARGET CELLS
#444RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use
#445RNA-EDITING OLIGONUCLEOTIDES AND USES THEREOF
#446SIRNA MOLECULE AGAINST HUMAN TENASCIN-C (TNC) AND A PHARMACEUTICAL COMPOSITION COMPRISING IT
#447COMPOUNDS AND METHODS FOR REDUCING PCDH19 EXPRESSION
#448Method for Treating Cyclophilin D Associated Diseases
#449COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION
#450COMPOSITION FOR CONTROLLING DNA DAMAGE REPAIR EFFICIENCY
#451SYSTEMS, METHODS, AND COMPOSITIONS FOR ALTERING THE EXPRESSION OF ENDOGENOUS CIRCULAR RNAS
#452LENTIVIRAL-BASED VECTORS AND RELATED SYSTEMS AND METHODS FOR EUKARYOTIC GENE EDITING
#453METHODS OF TREATING, AMELIORATING AND/OR PREVENTING POLYCYSTIC KIDNEY DISEASE AND POLYCYSTIC LIVER DISEASE
#454MODIFIED HETERONUCLEIC ACID CONTAINING MORPHOLINO NUCLEIC ACID
#455METHODS AND COMPOSITIONS FOR MODULATING APOLIPOPROTEIN (A) EXPRESSION
#456RNA MOLECULES FOR TREATING INSECTS
#457Conjugated Antisense Compounds and Their Use
#458POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF ANGPTL3, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#45917ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#460BBB-CROSSING LIPID LIGAND OF HETERO NUCLEIC ACID
#461RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use
#462Antisense oligonucleotides for the treatment of Stargardt disease
#463NOVEL TARGETS AGAINST OVARIAN CANCER
#464TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#465TRANSCRIPTIONALLY RECORDING CELL COMPOSITION AND METHOD FOR NON-INVASIVE ASSESSMENT OF GUT FUNCTION
#466SIRNA FOR INHIBITING ANGPTL3 GENE EXPRESSION AND USE THEREOF
#467PERSONALIZED CELLS, TISSUES, AND ORGANS FOR TRANSPLANTATION FROM A HUMANIZED, BESPOKE, DESIGNATED-PATHOGEN FREE, (NON-HUMAN) DONOR AND METHODS AND PRODUCTS RELATING TO SAME
#468COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#469COMPOSITIONS AND METHODS FOR MODULATING MYC TARGET PROTEIN 1
#470CARDIOPROTECTIVE HEART DISEASE THERAPIES
#471LPA-TARGETING SIRNA AND CONJUGATE
#472STEM CELL-DERIVED EXOSOMES FOR THE TREATMENT OF CORNEAL SCARRING
#473IONIZABLE CATIONIC LIPIDS FOR LIPID NANOPARTICLES
#474DETECTION ASSAYS
#475MODIFIED AAV CONSTRUCTS AND USES THEREOF
#476CHEMICALLY MODIFIED ANTISENSE OLIGONUCLEOTIDES (ASOS) AND COMPOSITIONS FOR RNA EDITING
#4775-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER
#478THE RARE CODON RECODING PLATFORM FOR NONCANONICAL AMINO ACIDS INCORPORATION IN MAMMALIAN CELLS
#479OLIGONUCLEOTIDES FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#480ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF
#481SUSTAINED RELEASE NUCLEIC ACID FORMULATIONS FOR TREATMENT OF PERIPHERAL NERVE DEMYELINATION
#482COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT FACTOR B
#483ROLE OF POLYPHOSPHATES IN NEUROLOGICAL DISORDERS
#484USE OF MYOSTATIN INHIBITOR FOR TREATING SPINAL MUSCULAR ATROPHY
#485COMPOSITIONS AND METHODS FOR REDUCING CELL THERAPY IMMUNOGENICITY
#486TREATMENTS FOR CHARCOT-MARIE-TOOTH DISEASE
#487POLYVALENT MOLECULE BASED LIPID NANOPARTICLES FOR NUCLEIC ACID DELIVERY
#488PLASMA piRNA COMBINATION FOR EARLY DIAGNOSIS OF GASTRIC CANCER AND APPLICATION THEREOF
#489AAV VECTORS FOR RETINAL AND CNS GENE THERAPY
#490TRANGENIC RODENTS FOR CELL LINE IDENTIFICATION AND ENRICHMENT
#491METHODS AND COMPOSITIONS FOR MODIFYING ROOT ARCHITECTURE IN PLANTS
#492MODULATION OF ABCB11 GENE TRANSCRIPTION USING ANTISENSE OLIGONUCLEOTIDES TARGETING REGULATORY RNAS
#493INHIBITION OF FOLLISTATIN
#494INHIBITORS OF EXPRESSION AND/OR FUNCTION
#495METHODS FOR REDUCING TAU EXPRESSION
#496CRISPR-CPF1-RELATED METHODS, COMPOSITIONS AND COMPONENTS FOR CANCER IMMUNOTHERAPY
#497COMPOSITIONS AND METHODS OF NUCLEIC ACID-TARGETING NUCLEIC ACIDS
#498NOVEL RNA-PROGRAMMABLE ENDONUCLEASE SYSTEMS AND USES THEREOF
#499RNA RECOGNITION COMPLEX AND USES THEREOF
#500METHODS AND COMPOSITIONS FOR TREATING FIBROSIS
#501Conjugated Antisense Compounds for Use in Therapy
#502Compositions and Methods for Modulating Cytokines
#503NUCLEIC ACID MOLECULE FOR REDUCTION OF PAPD5 AND PAPD7 mRNA FOR TREATING HEPATITIS B INFECTION
#504METHODS OF DELIVERING THERAPEUTIC AGENTS, AND LIPID COMPOSITIONS
#505METHODS AND COMPOSITIONS FOR MODULATING FIBRINOGEN
#506DNAZYMES FOR SENSING AND IMAGING TARGET MOLECULES
#507PRODUCTS AND COMPOSITIONS
#508MUCIN-5B (MUC5B) TARGETED SIRNA AND ANTISENSE OLIGONUCLEOTIDES AND METHODS OF USE THEREOF
#509CONJUGATES FOR TISSUE-SPECIFIC OLIGONUCLEOTIDE DELIVERY
#510NUCLEIC ACID FOR TRANSFECTION
#511PRODUCTS AND COMPOSITIONS
#512CHIRAL DESIGN
#513MICELLAR NANOPARTICLES AND USES THEREOF
#514RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF
#515ANTISENSE OLIGONUCLEOTIDE FOR TREATING MELANOMA
#516COMPOSITIONS FOR TREATING SYNGAP-1 RELATED NEURODEVELOPMENTAL DISORDERS
#517SEQUENCE DETERMINANTS OF DSRNA PROCESSING BY DICER
#518Facile Assembly of Soft Nanoarchitectures and Co-Loading of Hydrophilic and Hydrophobic Molecules via Flash Nanoprecipitation
#519GELATIN AND LIPIDOID GENETIC DELIVERY PARTICLE
#520COMPOSITIONS OF LIPID NANOPARTICLES FOR PLASMID DNA DELIVERY TO THE LIVER AND METHODS FOR PREPARING THE SAME
#521COMPOSITIONS AND METHODS FOR FACILITATING DELIVERY OF SYNTHETIC NUCLEIC ACIDS TO CELLS
#522METHODS FOR EVALUATION OF EXTRACELLULAR VESICLES
#523METHOD FOR DETECTING TARGET NUCLEIC ACID BY CLEAVING NON-NATURAL SEQUENCE USING CAS13 PROTEIN
#524TRANSCRIPTION ACTIVATORS AND PROGRAMMABLE TRANSCRIPTION ENGINEERING
#525CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#526NUCLEIC ACIDS ENCODING CRISPR-ASSOCIATED PROTEINS AND USES THEREOF
#527APTAMER AND RIBOZYME EQUILIBRIUM SHIFTING (ARES) RNA CIRCUITS AND USES THEREOF
#528Methods for Reducing Ataxin-2 Expression
#529COMPOSITIONS AND METHODS FOR SPLICING MODULATION OF UNC13A
#530REGULATION OF ARTIFICIAL MIRNAS BY ENDOGENOUS TISSUE-SPECIFIC MIRNAS AND METHODS OF USING THE SAME
#531STEREOSPECIFIC LINKAGES IN RNA EDITING OLIGONUCLEOTIDES
#532EDITING OLIGONUCLEOTIDE
#533CIRCULAR RNA CIRC-MAGI1 AND USES THEREOF
#534PROGRAMMABLE RECRUITMENT OF TRANSCRIPTION FACTORS TO ENDOGENOUS GENES
#535METHOD AND MOLECULES FOR REDUCING AXONAL TAU PROTEIN ACCUMULATION THROUGH BLOCKING OF HNRNP R-MEDIATED MAPT MRNA TRANSPORT FOR TREATMENT OF ALZHEIMER'S DISEASE
#536SINGLE-STRANDED LOOP OLIGONUCLEOTIDES
#537miRNA-BASED COMPOSITIONS AND METHODS OF USE THEREOF
#538COMPOSITIONS AND METHODS FOR MYOSIN HEAVY CHAIN BASE EDITING
#539REPROGRAMMABLE FANZOR POLYNUCLEOTIDES AND USES THEREOF
#540METHODS AND COMPOSITIONS OF VIRUS-LIKE PARTICLES OF CYTOPLASMIC TYPE CITRUS LEPROSIS VIRUS FOR NANOTECHNOLOGY APPLICATIONS
#541MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MUSCULAR DYSTROPHY
#542AMINOOXY CLICK CHEMISTRY (AOCC): A VERSATILE CONJUGATION APPROACH
#543METHOD OF SYNTHESIS OF AN IONIZABLE CATIONIC LIPID
#544NOVEL LIPIDS BASED ON OLIGO-y-GLUTAMIC ACID DERIVATIVES AND LIPID NANOPARTICLES CONTAINING THE SAME, AND USES THEREOF
#545Saponin Conjugates
#546RNAi Agents for Inhibiting Expression of Microtubule Associated Protein Tau (MAPT), Compositions Thereof, and Methods of Use
#547OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#548METHODS OF USING LONG NON-CODING RNA-8 (TROLL-8) AS A TARGET FOR CANCER DETECTION AND TREATMENT
#549TRANSGENE CASSETTES DESIGNED TO EXPRESS A HUMAN MECP2 GENE
#550RNA-BASED CONTROL OF POWDERY MILDEW
#551cGMP EXOSOME LOADED THERAPEUTICS FOR TREATING SICKLE CELL DISEASE
#552SYSTEMS TARGETING TMPRSS4 AND SLC34A2
#553COMPOUNDS AND METHODS FOR MODULATING ATXN1
#554ARTIFICIAL RNA MOLECULE
#555Nucleic acid regulation of SNCA
#556CERTAIN DUX4 INHIBITORS AND METHODS OF USE THEREOF
#557COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF PROTEIN LPA(APO(A))
#558ANTISENSE OLIGONUCLEOTIDE COMPLEX
#559METHODS AND COMPOSITIONS FOR INHIBITING MISMATCH REPAIR
#560MUC5AC-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR MODULATING MUCIN EXPRESSION
#561COMPOSITION AND METHOD FOR GENOME EDITING
#562MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#563NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#564COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION
#565COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#566MODIFIED IMMUNE CELL
#567ISOLATION OF ANTI-INFLAMMATORY NEUTROPHIL OR MONOCYTE SUBSET AND USE IN TREATING CARDIOVASCULAR DISEASES
#568DEFORMABLE NANO-SCALE VEHICLES (DNVS) FOR TRANS-BLOOD BRAIN BARRIER, TRANS-MUCOSAL, AND TRANSDERMAL DRUG DELIVERY
#569DIFFERENTIAL ALTERNATIVE SPLICING IN RELAPSED AND REFRACTORY DIFFUSE LARGE-B CELL LYMPHOMA PATIENTS RECEIVING CAR-T THERAPY
#570VARIANT RNAi
#571TARGETED TREATMENT OF SPLICEOPATHY-INDUCED NEUROLOGICAL DISORDERS
#572CHEMICALLY MODIFIED ANTISENSE OLIGONUCLEOTIDES (ASOS) AND COMPOSITIONS COMPRISING THE SAME FOR RNA EDITING
#573MODULATION OF SYNGAP1 GENE TRANSCRIPTION USING ANTISENSE OLIGONUCLEOTIDES TARGETING REGULATORY RNAS
#574STAT3 TARGETING OLIGONUCLEOTIDES AND USES THEREOF
#575DNAZYME SENSORS AND IMAGING PROBES FOR DETECTION OF METAL IONS AND METABOLITES IN CELLS
#576EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
#577IMPROVED OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES
#578LOCALIZATION OF TRANS-SPLICING NUCLEIC ACID MOLECULES TO AND WITHIN THE CELLULAR NUCLEUS
#579COMPOSITIONS FOR THE SILENCING OF snoRNAS AND METHODS OF USING SAME
#580METHODS FOR MODULATING HUMAN L1 RETROTRANSPOSONS RNA AND COMPOSITIONS FOR USE THEREIN
#581COMPOSITIONS AND METHODS FOR PROMOTING HOMOLOGY DIRECTED REPAIR
#582Compositions and Methods for RNA Editing
#583MIRNA COMBINATION FOR THE PREVENTION AND TREATMENT OF CANCER
#584COMPOSITIONS AND METHODS FOR TREATMENT OF KIDNEY DISEASE
#585Oligonucleotide Terminal Phosphate Derivatives and Method of Use
#586MAPT ANTISENSE OLIGONUCLEOTIDE
#587COMPOSITIONS AND METHODS FOR SPLICING MODULATION OF UNC13A
#588Compositions for Treatment of Polycystic Kidney Disease
#589Compounds and Methods for Modulating UBE3A-ATS
#590GENE THERAPY OF HIPPO SIGNALING IMPROVES HEART FUNCTION IN A CLINICALLY RELEVANT MODEL
#591ACTIN-BINDING LIM PROTEIN 3 (ABLIM3) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#592RNA COMPOSITIONS AND THERAPEUTIC METHODS THEREOF
#593ENHANCED HAMMERHEAD RIBOZYMES AND METHODS OF USE
#594TREATMENT OF CARDIOVASCULAR DISEASE
#595COMPOSITIONS FOR TARGETING FLI-1 AND METHODS OF USE THEREOF
#596CLUSTERIN OVEREXPRESSION IN ALZHEIMER’S DISEASE
#597Circular RNA Compositions and Methods
#598MINIMAL NEPHRIN PROMOTER
#599MODIFIED DOUBLE STRANDED OLIGONUCLEOTIDES
#600GENE-DRIVE IN DNA VIRUSES