ClassID:

109048

C12N15/113 - page 4 - CPC Classification

Classification description:

Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides

Recent Application in this class:
#901
20250152655
2025-05-15

EDIBLE PLANT-DERIVED NANOPARTICLES FOR REGULATION OF GUT MICROBIOTA

#902
20250152605
2025-05-15

METHOD AND DRUG FOR TREATING NEURONAL CEROID LIPOFUSCINOSIS

#903
20250152513
2025-05-15

METHOD FOR PREPARING LIPOSOMES

#904
20250146024
2025-05-08

Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription

#905
20250146005
2025-05-08

METHODS OF MAKING CIRCULAR RNA

#906
20250146004
2025-05-08

Materials and Methods for Treatment of Human Genetic Diseases Including Hemoglobinopathies

#907
20250145998
2025-05-08

COMPOSITIONS AND METHODS FOR GENE EDITING BY TARGETING TRANSFERRIN

#908
20250145997
2025-05-08

Antisense Nucleic Acids

#909
20250145996
2025-05-08

OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES

#910
20250145995
2025-05-08

MULTI-FUNCTIONAL COMBINATION OUTLINE TOOL

#911
20250145994
2025-05-08

COMPOSITIONS AND METHODS FOR TREATING CONDITIONS RELATED TO CELLULAR SENESCENCE

#912
20250145993
2025-05-08

ENHANCED EXPRESSION OF ALTERNATIVE SPLICED UROMODULIN FOR THERAPEUTICUSE

#913
20250145992
2025-05-08

OLIGONUCLEOTIDES WITH ETHYLENE GLYCOL MODIFICATION

#914
20250145991
2025-05-08

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#915
20250145990
2025-05-08

TRANS-SPLICING RNA (TSRNA)

#916
20250145966
2025-05-08

ENHANCED IMMUNE EFFECTOR CELLS AND USE THEREOF

#917
20250145952
2025-05-08

T CELLS WITH IMPROVED FUNCTIONALITY

#918
20250143624
2025-05-08

Ventricular Arrhythmias and Related Methods

#919
20250137892
2025-05-01

METHODS, COMPOSITIONS, AND DEVICES INVOLVING PSEUDOKNOT FORMATION

#920
20250137003
2025-05-01

ORGANELLE GENOME MODIFICATION USING POLYNUCLEOTIDE GUIDED ENDONUCLEASE

#921
20250136988
2025-05-01

ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF

#922
20250136987
2025-05-01

CHANNEL MODULATORS

#923
20250136986
2025-05-01

MODULATORS OF MALAT1 EXPRESSION

#924
20250136985
2025-05-01

miR-141-3p MODULATORS AND USES THEREOF

#925
20250136984
2025-05-01

OLIGONUCLEOTIDE AGONISTS TARGETING PROGRANULIN

#926
20250136983
2025-05-01

Composition and Methods for Modulating Nuclear Enriched Abundant Transcript 1 to Treat Cognitive Impairment

#927
20250136982
2025-05-01

MODULATION OF ALPHA SYNUCLEIN EXPRESSION

#928
20250136981
2025-05-01

COMPOSITIONS AND METHODS COMPRISING ENGINEERED SHORT NUCLEAR RNA (SNRNA)

#929
20250136980
2025-05-01

MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOPATHIES

#930
20250136979
2025-05-01

Methods and Compositions for Avoiding Off-Target Effects

#931
20250136978
2025-05-01

iRNA Compositions and Methods for Silencing ANGPTL4

#932
20250136977
2025-05-01

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF COMPLEMENT FACTOR B (CFB) IN A CELL

#933
20250136976
2025-05-01

USE OF ETV3 OR ETV6 INHIBITORS FOR BLOCKING THE DIFFERENTIATION OF MONOCYTES INTO DENDRITIC CELLS

#934
20250136942
2025-05-01

METHODS TO ACCELERATE STEM CELL DIFFERENTIATION TO CARDIOMYOCYTES

#935
20250136651
2025-05-01

RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT SYNDROME AND RELATED DISORDERS

#936
20250135036
2025-05-01

COMPOSITIONS FOR EDITING MECP2 TRANSCRIPTS AND METHODS THEREOF

#937
20250135015
2025-05-01

CELL-PENETRATING PEPTIDES FOR ANTISENSE DELIVERY

#938
20250134927
2025-05-01

COMPOSITIONS AND METHODS FOR TREATING OR PREVENTING AUTOIMMUNE DISEASES

#939
20250134920
2025-05-01

Treatment Of Myeloid Cell Dysfunction With Membrane Spanning 4-Domains A6A (MS4A6A) Inhibitors

#940
20250134919
2025-05-01

OPTIMIZED SEQUENCES FOR ENHANCED tRNA EXPRESSION OR/AND NONSENSE MUTATION SUPPRESSION

#941
20250129386
2025-04-24

NANOPARTICLE VECTOR FOR RNA SELF-DELIVERY, AND PREPARATION METHOD THEREFOR AND USE THEREOF

#942
20250129367
2025-04-24

METHODS AND COMPOSITIONS FOR TARGETED GENOMIC INSERTION

#943
20250129366
2025-04-24

Treatment Of Liver Disease Or Metabolic Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors

#944
20250129365
2025-04-24

COMPOUNDS AND METHODS FOR SKIPPING EXON 44 IN DUCHENNE MUSCULAR DYSTROPHY

#945
20250129363
2025-04-24

CRISPR/CAS SCREENING PLATFORM TO IDENTIFY GENETIC MODIFIERS OF TAU SEEDING OR AGGREGATION

#946
20250129170
2025-04-24

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#947
20250129147
2025-04-24

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#948
20250129137
2025-04-24

CD71 BINDING FIBRONECTIN TYPE III DOMAINS

#949
20250127809
2025-04-24

COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

#950
20250127719
2025-04-24

ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF

#951
20250127149
2025-04-24

MICRORNA INHIBITOR THERAPY IN SYSTEMIC LUPUS ERYTHEMATOSUS

#952
20250122537
2025-04-17

Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription

#953
20250122536
2025-04-17

NOVEL CAS9 ORTHOLOGS

#954
20250122500
2025-04-17

RNAi OLIGONUCLEOTIDE CONJUGATES

#955
20250122499
2025-04-17

ARTIFICIAL NUCLEIC ACIDS FOR RNA EDITING

#956
20250120914
2025-04-17

LIPID NANOPARTICLES

#957
20250116656
2025-04-10

OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION

#958
20250115923
2025-04-10

SIMULTANEOUS GENE EDITING AND HAPLOID INDUCTION

#959
20250115911
2025-04-10

SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE

#960
20250115910
2025-04-10

MODULATING THE CELLULAR STRESS RESPONSE

#961
20250115909
2025-04-10

COMPOUNDS FOR INHIBITING AMANZI

#962
20250115908
2025-04-10

METHOD OF INTERFERING WITH REPETITIVE RNA

#963
20250115907
2025-04-10

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA

#964
20250115906
2025-04-10

SCHWANN CELL-SPECIFIC PROMOTER

#965
20250115905
2025-04-10

Methods of Rescuing Stop Codons via Genetic Reassignment with ACE-tRNA

#966
20250115904
2025-04-10

EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6

#967
20250115877
2025-04-10

GENERATION OF INDUCED PLURIPOTENT CELLS BY CRISPR ACTIVATION

#968
20250114482
2025-04-10

THERAPEUTIC APPLICATIONS OF CPF1-BASED GENOME EDITING

#969
20250114478
2025-04-10

LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF

#970
20250114470
2025-04-10

THERAPY FOR POLYCYSTIC KIDNEY DISEASE

#971
20250114464
2025-04-10

PRE-MRNA SLICE MODULATING PEPTIDE-CONJUGATED ANTISENSE THERAPEUTICS FOR THE TREATMENT OF DISEASES

#972
20250114453
2025-04-10

METHODS FOR ENHANCING THERAPEUTIC EFFICACY OF ISOLATED CELLS FOR CELL THERAPY

#973
20250114306
2025-04-10

METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF

#974
20250113829
2025-04-10

HIGH MOLECULAR WEIGHT MODIFIED RNA COMPOSITIONS

#975
20250109409
2025-04-03

RIG1 Inhibition and Therapeutic Viral Protein Expression

#976
20250109399
2025-04-03

SIGNAL BOOST CASCADE ASSAY

#977
20250109398
2025-04-03

COMPOSITIONS FOR TREATING NEUROLOGICAL DISEASE

#978
20250109397
2025-04-03

RNA MOLECULE

#979
20250109396
2025-04-03

COMPOUNDS AND METHODS FOR MODULATING PROGRANULIN EXPRESSION

#980
20250109395
2025-04-03

S. PYOGENES CAS9 MUTANT GENES AND POLYPEPTIDES ENCODED BY SAME

#981
20250109164
2025-04-03

COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS

#982
20250108131
2025-04-03

TRIGGER NUCLEIC ACIDS AND RNA-BINDING PROTEINS FOR UPREGULATING GENE EXPRESSION

#983
20250108120
2025-04-03

COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES

#984
20250108067
2025-04-03

COMPOSITIONS FOR AQUACULTURING

#985
20250101463
2025-03-27

VECTOR-FREE INTRACELLULAR DELIVERY BY REVERSIBLE PERMEABILISATION

#986
20250101435
2025-03-27

COMPOSITIONS AND METHODS TO TREAT CANCER

#987
20250101426
2025-03-27

DEAMINASE-BASED RNA SENSORS

#988
20250101425
2025-03-27

NANOPARTICLES FUNCTIONALIZED WITH GENE EDITING TOOLS AND RELATED METHODS

#989
20250101424
2025-03-27

MIRNA CIRCUITS FOR CONTROLLED GENE EXPRESSION

#990
20250101423
2025-03-27

ADVANCED RNA TARGETING (ARNATAR)

#991
20250101422
2025-03-27

METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT

#992
20250101421
2025-03-27

OLIGONUCLEOTIDE MODULATORS ACTIVATING UTROPHIN EXPRESSION

#993
20250101420
2025-03-27

MODIFIED siRNA FOR SELECTIVELY INHIBITING EXPRESSION OF MUTANT FUS

#994
20250101419
2025-03-27

ALLELE SPECIFIC SPLICE SWITCHING OLIGONUCLEOTIDES TARGETING PSEUDOEXONS

#995
20250101418
2025-03-27

CHEMICALLY MODIFIED ANTISENSE OLIGONUCLEOTIDES (ASOS) AND COMPOSITIONS COMPRISING THE SAME FOR RNA EDITING

#996
20250101417
2025-03-27

Implantable Medical Device for the Delivery of a Nucleic Acid

#997
20250101383
2025-03-27

METHODS AND COMPOSITIONS FOR CARDIAC MODELS

#998
20250101093
2025-03-27

ANTI-IL-23 ANTIBODIES

#999
20250099603
2025-03-27

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA

#1000
20250099594
2025-03-27

TARGETED COMPOSITIONS

#1001
20250099566
2025-03-27

COMPOSITIONS AND METHODS FOR TREATING BACTERIAL DISEASE

#1002
20250099422
2025-03-27

COMPOSITIONS AND METHODS FOR TREATING ALLERGIC INFLAMMATORY CONDITIONS

#1003
20250099394
2025-03-27

LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF

#1004
20250092431
2025-03-20

Method for Regulating and Controlling Heterologous Synthetic Flavonoid Compound and Use Thereof

#1005
20250092402
2025-03-20

MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER

#1006
20250092399
2025-03-20

GENE THERAPY TARGETING THE NEONATAL FORM OF NAV1.5 FOR TREATING CANCER

#1007
20250092398
2025-03-20

POLYPEPTIDES USEFUL FOR GENE EDITING AND METHODS OF USE

#1008
20250092397
2025-03-20

RIBOZYME-ASSISTED CIRCULAR RNAS AND COMPOSITIONS AND METHODS OF USE THEREOF

#1009
20250092396
2025-03-20

Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors

#1010
20250092395
2025-03-20

A GLUN2D INHIBITOR FOR USE IN THE TREATMENT OR RELAPSE PREVENTION OF A DEPRESSIVE EPISODE

#1011
20250092394
2025-03-20

BANCR Compositions and Methods for Treating Disease

#1012
20250092393
2025-03-20

EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

#1013
20250092392
2025-03-20

ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATMENT OF NEURODEGENERATIVE DISORDERS

#1014
20250092391
2025-03-20

PROMOTERS FOR VIRAL-BASED GENE THERAPY

#1015
20250092390
2025-03-20

SYSTEMS, METHODS, AND COMPOSITIONS FOR SITE-SPECIFIC GENETIC ENGINEERING USING PROGRAMMABLE ADDITION VIA SITE-SPECIFIC TARGETING ELEMENTS (PASTE)

#1016
20250092389
2025-03-20

GUIDE RNA WITH CHEMICAL MODIFICATIONS

#1017
20250092388
2025-03-20

MICRORNA-33 INHIBITORS AND USE THEREOF IN THE TREATMENT OF PULMONARY FIBROSIS

#1018
20250092161
2025-03-20

PROMOTION SYSTEM FOR CELLULAR PROTEIN SYNTHESIS AND USE THEREOF

#1019
20250092072
2025-03-20

Trialkyne Linking Agents and Methods of Use

#1020
20250090685
2025-03-20

Cationic Hyperbranched Starch-based Gene Carrier, Preparation Method and Application Thereof

#1021
20250090588
2025-03-20

METHODS OF TREATING OR PREVENTING PREMATURE OVARIAN INSUFFICIENCY, POLYCYSTIC OVARY SYNDROME, OR INFERTILITY USING EXOSOMES OR MESENCHYMAL STEM CELLS

#1022
20250090569
2025-03-20

EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

#1023
20250090460
2025-03-20

Neurosome/Astrosome Compositions and Methods of Use

#1024
20250090197
2025-03-20

CANNULA SYSTEM AND USE THEREOF

#1025
20250084435
2025-03-13

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#1026
20250084414
2025-03-13

NONVIRAL VECTORS FOR GENE THERAPY

#1027
20250084413
2025-03-13

METHODS AND COMPOSITIONS TO REGULATE MAPT SPLICING FOR MODELING AND TREATMENT OF TAUOPATHIES

#1028
20250084412
2025-03-13

Antisense Nucleic Acids

#1029
20250084411
2025-03-13

Antisense Nucleic Acid

#1030
20250084390
2025-03-13

RECRUITMENT OF DNA POLYMERASE FOR TEMPLATED EDITING

#1031
20250084141
2025-03-13

RNA ENCODING A THERAPEUTIC PROTEIN

#1032
20250084137
2025-03-13

METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS

#1033
20250084030
2025-03-13

LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS

#1034
20250084029
2025-03-13

LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS

#1035
20250082766
2025-03-13

TREATMENT OF BRAIN TUMORS BY TARGETING THE CHOLESTEROL PATHWAY IN ASTROCYES

#1036
20250082685
2025-03-13

METHODS FOR ATTENUATING VIRAL INFECTION AND FOR TREATING LUNG INJURY

#1037
20250082682
2025-03-13

SYSTEMS OF ENGINEERED RECEPTORS TARGETING PSMA AND CA9

#1038
20250082679
2025-03-13

Method of Targeting Cells and Associated Compositions

#1039
20250075268
2025-03-06

CRISPR EFFECTOR SYSTEM BASED DIAGNOSTICS

#1040
20250075232
2025-03-06

NUCLEIC ACID-GUIDED NUCLEASES

#1041
20250075230
2025-03-06

WPRE MUTANT CONSTRUCTS, COMPOSITIONS, AND METHODS THEREOF

#1042
20250075215
2025-03-06

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND MOTOR BEHAVIOR

#1043
20250075214
2025-03-06

RNAi Agents for Inhibiting Expression of Inhibin Subunit Beta E (INHBE), Pharmaceutical Compositions Thereof, and Methods of Use

#1044
20250075213
2025-03-06

METHODS AND COMPOSITIONS FOR TREATING CARDIOMYOPATHY

#1045
20250075212
2025-03-06

L-RNA APTAMERS, RECOMBINANT POLYNUCLEOTIDES, AND USES THEREOF IN TREATING ALZHEIMERS DISEASE

#1046
20250075211
2025-03-06

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES

#1047
20250075210
2025-03-06

TARGETING THE YTHDF1/ARHGEF2 AXIS FOR CANCER TREATMENT

#1048
20250075209
2025-03-06

RNAS FOR COMPLEMENT INHIBITION

#1049
20250075208
2025-03-06

OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION

#1050
20250074977
2025-03-06

METHOD FOR IMPROVING WOUND HEALING

#1051
20250074933
2025-03-06

DOUBLE-STRANDED RNA HAVING NUCLEOTIDE ANALOG

#1052
20250074867
2025-03-06

NOVEL CATIONIC LIPID COMPOUNDS

#1053
20250074866
2025-03-06

MODIFIED AMINE LIPIDS

#1054
20250073342
2025-03-06

HYPERBRANCHED POLY(BETA-AMINO ESTER) FOR SIRNA DELIVERY AND GENE SILENCING

#1055
20250073257
2025-03-06

SMALL MOLECULE AND SIRNA INHIBITORS AGAINST LIPOCALIN-2

#1056
20250066855
2025-02-27

DETECTION OF GENETIC VARIANTS OF THE BETA-ADRENERGIC RECEPTOR PATHWAY FOR DETECTING AND TREATING RETINOPATHY OF PREMATURITY

#1057
20250066799
2025-02-27

UNNATURAL BASE PAIR COMPOSITIONS AND METHODS OF USE

#1058
20250066786
2025-02-27

ANGELMAN SYNDROME ANTISENSE TREATMENT

#1059
20250066785
2025-02-27

MODULATORS OF APOL1 EXPRESSION

#1060
20250066784
2025-02-27

THERAPEUTIC OLIGONUCLEOTIDES

#1061
20250066783
2025-02-27

POLYPEPTIDES USEFUL FOR GENE EDITING AND METHODS OF USE

#1062
20250066782
2025-02-27

Novel Retinitis Pigmentosa Treatment

#1063
20250066781
2025-02-27

METHODS FOR TREATING CONDITIONS AND DISEASES

#1064
20250066780
2025-02-27

OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING

#1065
20250066779
2025-02-27

Advanced RNA targeting (ARNATAR) for angiotensinogen

#1066
20250066778
2025-02-27

METHODS AND MATERIALS FOR TREATING HEART ATTACK

#1067
20250066777
2025-02-27

METHODS AND AGENTS FOR INCREASING RBM3 EXPRESSION

#1068
20250066776
2025-02-27

ANTISENSE OLIGOMERS FOR TREATMENT OF CHRONIC KIDNEY DISEASE

#1069
20250066775
2025-02-27

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

#1070
20250066741
2025-02-27

COMPOSITIONS AND METHODS FOR TRANSFER USING CER1

#1071
20250066496
2025-02-27

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#1072
20250066495
2025-02-27

Complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and method of delivering oligonucleotide to a subject

#1073
20250064980
2025-02-27

Materials and Methods for Treatment of Duchenne Muscular Dystrophy

#1074
20250064958
2025-02-27

AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENTS

#1075
20250064944
2025-02-27

MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF

#1076
20250064943
2025-02-27

ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1077
20250064940
2025-02-27

DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF

#1078
20250064938
2025-02-27

IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING

#1079
20250064936
2025-02-27

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#1080
20250064787
2025-02-27

Heterocyclic Carboxylate Compounds as Glycolate Oxidase Inhibitors

#1081
20250064752
2025-02-27

COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH

#1082
20250059576
2025-02-20

ANALYSIS OF NUCLEIC ACIDS ASSOCIATED WITH SINGLE CELLS USING NUCLEIC ACID BARCODES

#1083
20250059543
2025-02-20

METHODS AND COMPOSITIONS FOR TARGETED TRANS-SPLICING

#1084
20250059542
2025-02-20

CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1085
20250059541
2025-02-20

SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE

#1086
20250059540
2025-02-20

DOUBLE STRANDED RNA TARGETING ANGIOPOIETIN-LIKE 3 (ANGPTL-3) AND METHODS OF USE THEREOF

#1087
20250059539
2025-02-20

SGLT-2 TARGETING OLIGONUCLEOTIDES

#1088
20250059538
2025-02-20

COMPOSITIONS AND METHODS OF tRNA SILENCING

#1089
20250059537
2025-02-20

THERAPEUTIC OLIGONUCLEOTIDES HAVING AN INTER-NUCLEOSIDE AMIDE LINKAGE

#1090
20250059536
2025-02-20

TUNABLE REVERSIR TM COMPOUNDS

#1091
20250059535
2025-02-20

OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES

#1092
20250059534
2025-02-20

ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDITING WITH ENDOGENOUS ADENOSINE DEAMINASE ACTING ON RNA (ADAR)

#1093
20250059242
2025-02-20

METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS

#1094
20250057988
2025-02-20

Guide RNA That Targets A Mutant Human Guanylate Cyclase 2A Allele

#1095
20250057983
2025-02-20

COMPOSITION FOR PROMOTING MIGRATION OF ADULT STEM CELLS USING INCREASE IN EXPRESSION OF MIRNA

#1096
20250057870
2025-02-20

NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING NUCLEIC ACID, PREPARATION METHOD THEREFOR AND USE THEREOF

#1097
20250057836
2025-02-20

Compositions And Methods Targeting G12 Signaling For Bronchodilator Therapy

#1098
20250051788
2025-02-13

COMPOSITIONS FOR RNA-PROTEIN TETHERING AND METHODS OF USING

#1099
20250051777
2025-02-13

OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION

#1100
20250051776
2025-02-13

COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS ASSOCIATED WITH ARDS INDUCED PULMONARY FIBROSIS

#1101
20250051775
2025-02-13

THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS

#1102
20250051774
2025-02-13

DIRECT PRODUCTION OF SIRNAS IN SACCHAROMYCES BOULARDII AND PACKAGING IN EXTRACELLULAR VESICLES (EVs) FOR TARGETED GENE SILENCING

#1103
20250051773
2025-02-13

DNAZYME AND USE THEREOF

#1104
20250051772
2025-02-13

Antisense Oligonucleotide for Targeting Progranulin

#1105
20250051771
2025-02-13

MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF

#1106
20250051770
2025-02-13

COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS

#1107
20250051769
2025-02-13

ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA

#1108
20250051768
2025-02-13

NON-CODING RNA-MEDIATED NEUROLOGICAL DISEASE TREATMENT

#1109
20250051767
2025-02-13

iRNA Compositions and Methods for Silencing MYLIP

#1110
20250051766
2025-02-13

TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE TRANSCRIPTS

#1111
20250051765
2025-02-13

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1112
20250051424
2025-02-13

COMPOSITIONS AND METHODS FOR REGULATING PRODUCTION OF AN ANTIBODY LIKE PROTEIN AND RIBONUCLEIC ACID

#1113
20250051393
2025-02-13

COMPOSITIONS AND METHODS FOR MODULATING INTERFERON REGULATORY FACTOR-5 (IRF-5) ACTIVITY

#1114
20250049895
2025-02-13

TREATING & PREVENTING E COLI INFECTIONS

#1115
20250043291
2025-02-06

TRANSMISSIBLE ELEMENTS COMPRISING PATHWAY MODIFICATION SYSTEMS AND EXOGENOUS NUCLEIC ACIDS FOR THE PRODUCTION OF MOLECULES OF INTEREST

#1116
20250043288
2025-02-06

PRODUCTS AND COMPOSITIONS

#1117
20250043287
2025-02-06

SYNTHETIC MEMORY WITH INTERCEPTING RECOMBINASE FUNCTION

#1118
20250043286
2025-02-06

METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE

#1119
20250043285
2025-02-06

Mammalian ATG8 Proteins and ATG9A Direct Sealing of Autophagosomal Membranes

#1120
20250043284
2025-02-06

OLIGONUCLEOTIDES FOR SNCA MODULATION

#1121
20250043283
2025-02-06

PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS VIA FAST-FLOW SYNTHESIS

#1122
20250043282
2025-02-06

ATTENUATED ORTHOMYXOVIRUS-BASED VECTOR PLATFORM

#1123
20250043281
2025-02-06

TREATMENT OF FGG RELATED DISEASES AND DISORDERS

#1124
20250043280
2025-02-06

ANTISENSE OLIGONUCLEOTIDE FOR USE IN THE TREATMENT OF PSORIASIS-INDUCED ITCHING AND PHOSPHOLIPID VESICLE COMPRISING SAID OLIGONUCLEOTIDE

#1125
20250043279
2025-02-06

SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1126
20250042975
2025-02-06

NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO

#1127
20250042933
2025-02-06

ANTISENSE NUCLEIC ACIDS

#1128
20250041440
2025-02-06

COMPOSITIONS AND METHODS FOR PREVENTION OR REDUCTION OF CARPA

#1129
20250041423
2025-02-06

EXTRACTION OF PLANT SOURCE "MEDICINAL SOUP" AND MANUAL PREPARATION OF "HERBAL MEDICINE" AND RELATED PRODUCTS

#1130
20250040522
2025-02-06

MUTANT MYOCILIN DISEASE MODEL AND USES THEREOF

#1131
20250034572
2025-01-30

MODIFIED DOUBLE-STRANDED RNA AGENTS

#1132
20250034571
2025-01-30

NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY

#1133
20250034570
2025-01-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1134
20250034569
2025-01-30

ANTISENSE OLIGONUCLEOTIDE DRUG TARGETS

#1135
20250034568
2025-01-30

CONSTRUCTS COMPRISING TANDEM MICRORNA-ADAPTED SHORT HAIRPIN RNA (SHMIR) FOR INCREASING FETAL HEMOGLOBIN

#1136
20250034567
2025-01-30

CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1137
20250034566
2025-01-30

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#1138
20250034565
2025-01-30

GLYCAN CONJUGATE COMPOSITIONS AND METHODS

#1139
20250034564
2025-01-30

Methods and Compositions for ADAR-Mediated Editing

#1140
20250034563
2025-01-30

Methods and Compositions for ADAR-Mediated Editing

#1141
20250034562
2025-01-30

COMPOSITIONS AND METHODS FOR IMPROVING THE EFFICACY OF CAS9-BASED KNOCK-IN STRATEGIES

#1142
20250034561
2025-01-30

Novel Compositions for Conjugating Oligonucleotides and Carbohydrates

#1143
20250032628
2025-01-30

TARGETED VESICLE COMPOSITIONS AND METHODS

#1144
20250032622
2025-01-30

COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES

#1145
20250032459
2025-01-30

METHOD FOR TREATING NEURODEGENERATIVE DISEASES

#1146
20250027937
2025-01-23

DNA mapping and sequencing on linearized DNA molecules

#1147
20250027111
2025-01-23

TEMPERATURE-BASED TRANSIENT DELIVERY OF NUCLEIC ACIDS AND PROTEINS TO CELLS AND TISSUES

#1148
20250027107
2025-01-23

DNA COMPOSITIONS AND RELATED METHODS

#1149
20250027105
2025-01-23

COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY

#1150
20250027095
2025-01-23

Target gene expression control system comprising dxCas9 and CRP derivative and preparation method therefor

#1151
20250027086
2025-01-23

COMPOSITIONS AND METHODS FOR TREATMENT OF CANCERS USING MODIFIED siRNA-GEM AGENTS

#1152
20250027085
2025-01-23

COMPOSITIONS AND METHODS FOR TREATING ALZHEIMER'S DISEASE UTILIZING A TRANSCRIPTIONAL MASTER REGULATOR OF THE RETROMER COMPLEX

#1153
20250027084
2025-01-23

COMPOSITIONS FOR INHIBITING DIPEPTIDE REPEAT PROTEIN-RIBOSOMAL RNA INTERACTION AND USES THEREOF

#1154
20250027083
2025-01-23

USE OF MIRNA-2911 MOLECULE AS NUCLEIC ACID STABILIZER

#1155
20250027082
2025-01-23

STAGGERED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS

#1156
20250027081
2025-01-23

METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION

#1157
20250027080
2025-01-23

COMPLEMENT FACTOR B (CFB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1158
20250027079
2025-01-23

USE OF FANA ANTISENSE OLIGONUCLEOTIDES FOR THE PREVENTION AND MANAGEMENT OF HUANGLONGBING AND ZEBRA CHIP DISEASES

#1159
20250027065
2025-01-23

ENGINEERED NUCLEASES THAT TARGET HUMAN AND CANINE FACTOR VIII GENES AS A TREATMENT FOR HEMOPHILIA A

#1160
20250027054
2025-01-23

Compositions And Methods For Differentiation Of Human Pluripotent Stem Cells Into Desired Cell Types

#1161
20250025570
2025-01-23

MUSCLE TARGETING COMPLEXES FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#1162
20250025569
2025-01-23

TISSUE-SPECIFIC IMAGING AND THERAPEUTIC AGENTS TARGETING PROTEINS EXPRESSED ON MUSCLE CELL SURFACE

#1163
20250025509
2025-01-23

MESENCHYMAL STROMAL CELL DELIVERY VIA CARDIOPULMONARY BYPASS PROVIDES NEUROPROTECTION

#1164
20250025487
2025-01-23

THERAPEUTIC NUCLEIC ACIDS AND METHODS OF USE THEREOF

#1165
20250025486
2025-01-23

ANTICANCER COMPOSITIONS AND METHODS FOR MAKING AND USING THEM

#1166
20250019763
2025-01-16

HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS

#1167
20250019706
2025-01-16

Deaminase-Based RNA Sensors

#1168
20250019705
2025-01-16

PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING TARGET CANCER INCLUDING BRCA-SPECIFIC siRNA AS ACTIVE INGREDIENT

#1169
20250019704
2025-01-16

ANTITUMORAL COMPOSITION

#1170
20250019703
2025-01-16

PHARMACEUTICAL COMPOSITION FOR PREVENTION OR TREATMENT OF BLOOD CANCER COMPRISING SURF4 INHIBITOR

#1171
20250019702
2025-01-16

GATA4-TARGETED THERAPEUTICS FOR TREATMENT OF CARDIAC HYPERTROPHY

#1172
20250019701
2025-01-16

TREATMENT FOR INFLAMMATORY DISEASE

#1173
20250019700
2025-01-16

TREATING CHEMORESISTANT FORMS OF LEUKEMIA AND OTHER CANCERS THAT OVEREXPRESS RNA BINDING PROTEIN FXR1

#1174
20250019699
2025-01-16

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE

#1175
20250019698
2025-01-16

IRNA COMPOSITIONS AND METHODS FOR SILENCING COMPLEMENT COMPONENT 3 (C3)

#1176
20250019697
2025-01-16

MODIFIED U6 PROMOTER SYSTEM FOR TISSUE SPECIFIC EXPRESSION

#1177
20250019696
2025-01-16

USE OF GANODERMA FUNGAL RNA MOLECULES, DRUG, DRUG COMPOSITION AND DELIVERY CARRIER

#1178
20250019668
2025-01-16

ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV)

#1179
20250018050
2025-01-16

DOSING OF MUSCLE TARGETING COMPLEXES FOR TREATING DYSTROPHINOPATHIES

#1180
20250018045
2025-01-16

LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY

#1181
20250018030
2025-01-16

PHARMACEUTICAL COMPOSITION FOR PROMOTING CANCER IMMUNOTHERAPY AND METHOD FOR PROMOTING CANCER IMMUNOTHERAPY

#1182
20250017953
2025-01-16

LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1183
20250017220
2025-01-16

YEAST STRAIN FOR MOSQUITO MANAGEMENT

#1184
20250011785
2025-01-09

Compositions and Methods for Modulating Single Stranded DNA Regions that Catalyze Enzymatic Reactions

#1185
20250011784
2025-01-09

RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS

#1186
20250011783
2025-01-09

GENE THERAPY FOR NEURODEGENERATIVE DISORDERS

#1187
20250011782
2025-01-09

ARTIFICIAL YEAST PROMOTER REGIONS

#1188
20250011781
2025-01-09

METHODS AND COMPOSITIONS TARGETING NUCLEUS ACCUMBENS-ASSOCIATED PROTEIN-1 FOR TREATMENT OF AUTOIMMUNE DISORDERS AND CANCERS

#1189
20250011780
2025-01-09

COMPOSITIONS OF HUMAN HEART DERIVED EXTRACELLULAR VESICLES AND USES THEREOF

#1190
20250011779
2025-01-09

COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS

#1191
20250011778
2025-01-09

APP iRNA Compositions and Methods of Use Thereof for Treating or Preventing Diseases Characterized by Enlarged Endosomes

#1192
20250011777
2025-01-09

DELIVERY OF ANITSENSE OLIGOMERS BY MIRROR IMAGE PEPTIDES

#1193
20250011776
2025-01-09

HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1194
20250011775
2025-01-09

Engineered Guide RNAs and Polynucleotides

#1195
20250011774
2025-01-09

ANTISENSE COMPOUNDS AND METHODS FOR TARGETING CUG REPEATS

#1196
20250011773
2025-01-09

COMPOSITIONS AND METHODS FOR TREATING TDP-43 PROTEINOPATHY

#1197
20250011772
2025-01-09

NEURODEGENERATIVE DISORDERS

#1198
20250011756
2025-01-09

METHODS OF EDITING WITH ENGINEERED CLASS 2 TYPE V CRISPR SYSTEMS

#1199
20250011404
2025-01-09

TARGETING APOE ENHANCES T-CELL KILLING IN CANCER IMMUNOTHERAPY

#1200
20250011359
2025-01-09

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME