109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
EDIBLE PLANT-DERIVED NANOPARTICLES FOR REGULATION OF GUT MICROBIOTA
#902METHOD AND DRUG FOR TREATING NEURONAL CEROID LIPOFUSCINOSIS
#903METHOD FOR PREPARING LIPOSOMES
#904Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#905METHODS OF MAKING CIRCULAR RNA
#906Materials and Methods for Treatment of Human Genetic Diseases Including Hemoglobinopathies
#907COMPOSITIONS AND METHODS FOR GENE EDITING BY TARGETING TRANSFERRIN
#908Antisense Nucleic Acids
#909OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES
#910MULTI-FUNCTIONAL COMBINATION OUTLINE TOOL
#911COMPOSITIONS AND METHODS FOR TREATING CONDITIONS RELATED TO CELLULAR SENESCENCE
#912ENHANCED EXPRESSION OF ALTERNATIVE SPLICED UROMODULIN FOR THERAPEUTICUSE
#913OLIGONUCLEOTIDES WITH ETHYLENE GLYCOL MODIFICATION
#914EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#915TRANS-SPLICING RNA (TSRNA)
#916ENHANCED IMMUNE EFFECTOR CELLS AND USE THEREOF
#917T CELLS WITH IMPROVED FUNCTIONALITY
#918Ventricular Arrhythmias and Related Methods
#919METHODS, COMPOSITIONS, AND DEVICES INVOLVING PSEUDOKNOT FORMATION
#920ORGANELLE GENOME MODIFICATION USING POLYNUCLEOTIDE GUIDED ENDONUCLEASE
#921ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF
#922CHANNEL MODULATORS
#923MODULATORS OF MALAT1 EXPRESSION
#924miR-141-3p MODULATORS AND USES THEREOF
#925OLIGONUCLEOTIDE AGONISTS TARGETING PROGRANULIN
#926Composition and Methods for Modulating Nuclear Enriched Abundant Transcript 1 to Treat Cognitive Impairment
#927MODULATION OF ALPHA SYNUCLEIN EXPRESSION
#928COMPOSITIONS AND METHODS COMPRISING ENGINEERED SHORT NUCLEAR RNA (SNRNA)
#929MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOPATHIES
#930Methods and Compositions for Avoiding Off-Target Effects
#931iRNA Compositions and Methods for Silencing ANGPTL4
#932NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF COMPLEMENT FACTOR B (CFB) IN A CELL
#933USE OF ETV3 OR ETV6 INHIBITORS FOR BLOCKING THE DIFFERENTIATION OF MONOCYTES INTO DENDRITIC CELLS
#934METHODS TO ACCELERATE STEM CELL DIFFERENTIATION TO CARDIOMYOCYTES
#935RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT SYNDROME AND RELATED DISORDERS
#936COMPOSITIONS FOR EDITING MECP2 TRANSCRIPTS AND METHODS THEREOF
#937CELL-PENETRATING PEPTIDES FOR ANTISENSE DELIVERY
#938COMPOSITIONS AND METHODS FOR TREATING OR PREVENTING AUTOIMMUNE DISEASES
#939Treatment Of Myeloid Cell Dysfunction With Membrane Spanning 4-Domains A6A (MS4A6A) Inhibitors
#940OPTIMIZED SEQUENCES FOR ENHANCED tRNA EXPRESSION OR/AND NONSENSE MUTATION SUPPRESSION
#941NANOPARTICLE VECTOR FOR RNA SELF-DELIVERY, AND PREPARATION METHOD THEREFOR AND USE THEREOF
#942METHODS AND COMPOSITIONS FOR TARGETED GENOMIC INSERTION
#943Treatment Of Liver Disease Or Metabolic Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors
#944COMPOUNDS AND METHODS FOR SKIPPING EXON 44 IN DUCHENNE MUSCULAR DYSTROPHY
#945CRISPR/CAS SCREENING PLATFORM TO IDENTIFY GENETIC MODIFIERS OF TAU SEEDING OR AGGREGATION
#946EPO RECEPTOR AGONISTS AND ANTAGONISTS
#947EPO RECEPTOR AGONISTS AND ANTAGONISTS
#948CD71 BINDING FIBRONECTIN TYPE III DOMAINS
#949COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#950ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF
#951MICRORNA INHIBITOR THERAPY IN SYSTEMIC LUPUS ERYTHEMATOSUS
#952Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription
#953NOVEL CAS9 ORTHOLOGS
#954RNAi OLIGONUCLEOTIDE CONJUGATES
#955ARTIFICIAL NUCLEIC ACIDS FOR RNA EDITING
#956LIPID NANOPARTICLES
#957OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#958SIMULTANEOUS GENE EDITING AND HAPLOID INDUCTION
#959SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE
#960MODULATING THE CELLULAR STRESS RESPONSE
#961COMPOUNDS FOR INHIBITING AMANZI
#962METHOD OF INTERFERING WITH REPETITIVE RNA
#963COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA
#964SCHWANN CELL-SPECIFIC PROMOTER
#965Methods of Rescuing Stop Codons via Genetic Reassignment with ACE-tRNA
#966EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
#967GENERATION OF INDUCED PLURIPOTENT CELLS BY CRISPR ACTIVATION
#968THERAPEUTIC APPLICATIONS OF CPF1-BASED GENOME EDITING
#969LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF
#970THERAPY FOR POLYCYSTIC KIDNEY DISEASE
#971PRE-MRNA SLICE MODULATING PEPTIDE-CONJUGATED ANTISENSE THERAPEUTICS FOR THE TREATMENT OF DISEASES
#972METHODS FOR ENHANCING THERAPEUTIC EFFICACY OF ISOLATED CELLS FOR CELL THERAPY
#973METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF
#974HIGH MOLECULAR WEIGHT MODIFIED RNA COMPOSITIONS
#975RIG1 Inhibition and Therapeutic Viral Protein Expression
#976SIGNAL BOOST CASCADE ASSAY
#977COMPOSITIONS FOR TREATING NEUROLOGICAL DISEASE
#978RNA MOLECULE
#979COMPOUNDS AND METHODS FOR MODULATING PROGRANULIN EXPRESSION
#980S. PYOGENES CAS9 MUTANT GENES AND POLYPEPTIDES ENCODED BY SAME
#981COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS
#982TRIGGER NUCLEIC ACIDS AND RNA-BINDING PROTEINS FOR UPREGULATING GENE EXPRESSION
#983COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#984COMPOSITIONS FOR AQUACULTURING
#985VECTOR-FREE INTRACELLULAR DELIVERY BY REVERSIBLE PERMEABILISATION
#986COMPOSITIONS AND METHODS TO TREAT CANCER
#987DEAMINASE-BASED RNA SENSORS
#988NANOPARTICLES FUNCTIONALIZED WITH GENE EDITING TOOLS AND RELATED METHODS
#989MIRNA CIRCUITS FOR CONTROLLED GENE EXPRESSION
#990ADVANCED RNA TARGETING (ARNATAR)
#991METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#992OLIGONUCLEOTIDE MODULATORS ACTIVATING UTROPHIN EXPRESSION
#993MODIFIED siRNA FOR SELECTIVELY INHIBITING EXPRESSION OF MUTANT FUS
#994ALLELE SPECIFIC SPLICE SWITCHING OLIGONUCLEOTIDES TARGETING PSEUDOEXONS
#995CHEMICALLY MODIFIED ANTISENSE OLIGONUCLEOTIDES (ASOS) AND COMPOSITIONS COMPRISING THE SAME FOR RNA EDITING
#996Implantable Medical Device for the Delivery of a Nucleic Acid
#997METHODS AND COMPOSITIONS FOR CARDIAC MODELS
#998ANTI-IL-23 ANTIBODIES
#999MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA
#1000TARGETED COMPOSITIONS
#1001COMPOSITIONS AND METHODS FOR TREATING BACTERIAL DISEASE
#1002COMPOSITIONS AND METHODS FOR TREATING ALLERGIC INFLAMMATORY CONDITIONS
#1003LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF
#1004Method for Regulating and Controlling Heterologous Synthetic Flavonoid Compound and Use Thereof
#1005MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER
#1006GENE THERAPY TARGETING THE NEONATAL FORM OF NAV1.5 FOR TREATING CANCER
#1007POLYPEPTIDES USEFUL FOR GENE EDITING AND METHODS OF USE
#1008RIBOZYME-ASSISTED CIRCULAR RNAS AND COMPOSITIONS AND METHODS OF USE THEREOF
#1009Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors
#1010A GLUN2D INHIBITOR FOR USE IN THE TREATMENT OR RELAPSE PREVENTION OF A DEPRESSIVE EPISODE
#1011BANCR Compositions and Methods for Treating Disease
#1012EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#1013ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATMENT OF NEURODEGENERATIVE DISORDERS
#1014PROMOTERS FOR VIRAL-BASED GENE THERAPY
#1015SYSTEMS, METHODS, AND COMPOSITIONS FOR SITE-SPECIFIC GENETIC ENGINEERING USING PROGRAMMABLE ADDITION VIA SITE-SPECIFIC TARGETING ELEMENTS (PASTE)
#1016GUIDE RNA WITH CHEMICAL MODIFICATIONS
#1017MICRORNA-33 INHIBITORS AND USE THEREOF IN THE TREATMENT OF PULMONARY FIBROSIS
#1018PROMOTION SYSTEM FOR CELLULAR PROTEIN SYNTHESIS AND USE THEREOF
#1019Trialkyne Linking Agents and Methods of Use
#1020Cationic Hyperbranched Starch-based Gene Carrier, Preparation Method and Application Thereof
#1021METHODS OF TREATING OR PREVENTING PREMATURE OVARIAN INSUFFICIENCY, POLYCYSTIC OVARY SYNDROME, OR INFERTILITY USING EXOSOMES OR MESENCHYMAL STEM CELLS
#1022EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#1023Neurosome/Astrosome Compositions and Methods of Use
#1024CANNULA SYSTEM AND USE THEREOF
#1025TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#1026NONVIRAL VECTORS FOR GENE THERAPY
#1027METHODS AND COMPOSITIONS TO REGULATE MAPT SPLICING FOR MODELING AND TREATMENT OF TAUOPATHIES
#1028Antisense Nucleic Acids
#1029Antisense Nucleic Acid
#1030RECRUITMENT OF DNA POLYMERASE FOR TEMPLATED EDITING
#1031RNA ENCODING A THERAPEUTIC PROTEIN
#1032METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS
#1033LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS
#1034LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS
#1035TREATMENT OF BRAIN TUMORS BY TARGETING THE CHOLESTEROL PATHWAY IN ASTROCYES
#1036METHODS FOR ATTENUATING VIRAL INFECTION AND FOR TREATING LUNG INJURY
#1037SYSTEMS OF ENGINEERED RECEPTORS TARGETING PSMA AND CA9
#1038Method of Targeting Cells and Associated Compositions
#1039CRISPR EFFECTOR SYSTEM BASED DIAGNOSTICS
#1040NUCLEIC ACID-GUIDED NUCLEASES
#1041WPRE MUTANT CONSTRUCTS, COMPOSITIONS, AND METHODS THEREOF
#1042COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND MOTOR BEHAVIOR
#1043RNAi Agents for Inhibiting Expression of Inhibin Subunit Beta E (INHBE), Pharmaceutical Compositions Thereof, and Methods of Use
#1044METHODS AND COMPOSITIONS FOR TREATING CARDIOMYOPATHY
#1045L-RNA APTAMERS, RECOMBINANT POLYNUCLEOTIDES, AND USES THEREOF IN TREATING ALZHEIMERS DISEASE
#1046TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES
#1047TARGETING THE YTHDF1/ARHGEF2 AXIS FOR CANCER TREATMENT
#1048RNAS FOR COMPLEMENT INHIBITION
#1049OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION
#1050METHOD FOR IMPROVING WOUND HEALING
#1051DOUBLE-STRANDED RNA HAVING NUCLEOTIDE ANALOG
#1052NOVEL CATIONIC LIPID COMPOUNDS
#1053MODIFIED AMINE LIPIDS
#1054HYPERBRANCHED POLY(BETA-AMINO ESTER) FOR SIRNA DELIVERY AND GENE SILENCING
#1055SMALL MOLECULE AND SIRNA INHIBITORS AGAINST LIPOCALIN-2
#1056DETECTION OF GENETIC VARIANTS OF THE BETA-ADRENERGIC RECEPTOR PATHWAY FOR DETECTING AND TREATING RETINOPATHY OF PREMATURITY
#1057UNNATURAL BASE PAIR COMPOSITIONS AND METHODS OF USE
#1058ANGELMAN SYNDROME ANTISENSE TREATMENT
#1059MODULATORS OF APOL1 EXPRESSION
#1060THERAPEUTIC OLIGONUCLEOTIDES
#1061POLYPEPTIDES USEFUL FOR GENE EDITING AND METHODS OF USE
#1062Novel Retinitis Pigmentosa Treatment
#1063METHODS FOR TREATING CONDITIONS AND DISEASES
#1064OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING
#1065Advanced RNA targeting (ARNATAR) for angiotensinogen
#1066METHODS AND MATERIALS FOR TREATING HEART ATTACK
#1067METHODS AND AGENTS FOR INCREASING RBM3 EXPRESSION
#1068ANTISENSE OLIGOMERS FOR TREATMENT OF CHRONIC KIDNEY DISEASE
#1069OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#1070COMPOSITIONS AND METHODS FOR TRANSFER USING CER1
#1071MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#1072Complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and method of delivering oligonucleotide to a subject
#1073Materials and Methods for Treatment of Duchenne Muscular Dystrophy
#1074AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENTS
#1075MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF
#1076ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1077DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF
#1078IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#1079COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#1080Heterocyclic Carboxylate Compounds as Glycolate Oxidase Inhibitors
#1081COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH
#1082ANALYSIS OF NUCLEIC ACIDS ASSOCIATED WITH SINGLE CELLS USING NUCLEIC ACID BARCODES
#1083METHODS AND COMPOSITIONS FOR TARGETED TRANS-SPLICING
#1084CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1085SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE
#1086DOUBLE STRANDED RNA TARGETING ANGIOPOIETIN-LIKE 3 (ANGPTL-3) AND METHODS OF USE THEREOF
#1087SGLT-2 TARGETING OLIGONUCLEOTIDES
#1088COMPOSITIONS AND METHODS OF tRNA SILENCING
#1089THERAPEUTIC OLIGONUCLEOTIDES HAVING AN INTER-NUCLEOSIDE AMIDE LINKAGE
#1090TUNABLE REVERSIR TM COMPOUNDS
#1091OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#1092ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDITING WITH ENDOGENOUS ADENOSINE DEAMINASE ACTING ON RNA (ADAR)
#1093METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS
#1094Guide RNA That Targets A Mutant Human Guanylate Cyclase 2A Allele
#1095COMPOSITION FOR PROMOTING MIGRATION OF ADULT STEM CELLS USING INCREASE IN EXPRESSION OF MIRNA
#1096NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING NUCLEIC ACID, PREPARATION METHOD THEREFOR AND USE THEREOF
#1097Compositions And Methods Targeting G12 Signaling For Bronchodilator Therapy
#1098COMPOSITIONS FOR RNA-PROTEIN TETHERING AND METHODS OF USING
#1099OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
#1100COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS ASSOCIATED WITH ARDS INDUCED PULMONARY FIBROSIS
#1101THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#1102DIRECT PRODUCTION OF SIRNAS IN SACCHAROMYCES BOULARDII AND PACKAGING IN EXTRACELLULAR VESICLES (EVs) FOR TARGETED GENE SILENCING
#1103DNAZYME AND USE THEREOF
#1104Antisense Oligonucleotide for Targeting Progranulin
#1105MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF
#1106COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS
#1107ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA
#1108NON-CODING RNA-MEDIATED NEUROLOGICAL DISEASE TREATMENT
#1109iRNA Compositions and Methods for Silencing MYLIP
#1110TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE TRANSCRIPTS
#1111APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1112COMPOSITIONS AND METHODS FOR REGULATING PRODUCTION OF AN ANTIBODY LIKE PROTEIN AND RIBONUCLEIC ACID
#1113COMPOSITIONS AND METHODS FOR MODULATING INTERFERON REGULATORY FACTOR-5 (IRF-5) ACTIVITY
#1114TREATING & PREVENTING E COLI INFECTIONS
#1115TRANSMISSIBLE ELEMENTS COMPRISING PATHWAY MODIFICATION SYSTEMS AND EXOGENOUS NUCLEIC ACIDS FOR THE PRODUCTION OF MOLECULES OF INTEREST
#1116PRODUCTS AND COMPOSITIONS
#1117SYNTHETIC MEMORY WITH INTERCEPTING RECOMBINASE FUNCTION
#1118METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#1119Mammalian ATG8 Proteins and ATG9A Direct Sealing of Autophagosomal Membranes
#1120OLIGONUCLEOTIDES FOR SNCA MODULATION
#1121PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS VIA FAST-FLOW SYNTHESIS
#1122ATTENUATED ORTHOMYXOVIRUS-BASED VECTOR PLATFORM
#1123TREATMENT OF FGG RELATED DISEASES AND DISORDERS
#1124ANTISENSE OLIGONUCLEOTIDE FOR USE IN THE TREATMENT OF PSORIASIS-INDUCED ITCHING AND PHOSPHOLIPID VESICLE COMPRISING SAID OLIGONUCLEOTIDE
#1125SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1126NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO
#1127ANTISENSE NUCLEIC ACIDS
#1128COMPOSITIONS AND METHODS FOR PREVENTION OR REDUCTION OF CARPA
#1129EXTRACTION OF PLANT SOURCE "MEDICINAL SOUP" AND MANUAL PREPARATION OF "HERBAL MEDICINE" AND RELATED PRODUCTS
#1130MUTANT MYOCILIN DISEASE MODEL AND USES THEREOF
#1131MODIFIED DOUBLE-STRANDED RNA AGENTS
#1132NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
#1133STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1134ANTISENSE OLIGONUCLEOTIDE DRUG TARGETS
#1135CONSTRUCTS COMPRISING TANDEM MICRORNA-ADAPTED SHORT HAIRPIN RNA (SHMIR) FOR INCREASING FETAL HEMOGLOBIN
#1136CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1137COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#1138GLYCAN CONJUGATE COMPOSITIONS AND METHODS
#1139Methods and Compositions for ADAR-Mediated Editing
#1140Methods and Compositions for ADAR-Mediated Editing
#1141COMPOSITIONS AND METHODS FOR IMPROVING THE EFFICACY OF CAS9-BASED KNOCK-IN STRATEGIES
#1142Novel Compositions for Conjugating Oligonucleotides and Carbohydrates
#1143TARGETED VESICLE COMPOSITIONS AND METHODS
#1144COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#1145METHOD FOR TREATING NEURODEGENERATIVE DISEASES
#1146DNA mapping and sequencing on linearized DNA molecules
#1147TEMPERATURE-BASED TRANSIENT DELIVERY OF NUCLEIC ACIDS AND PROTEINS TO CELLS AND TISSUES
#1148DNA COMPOSITIONS AND RELATED METHODS
#1149COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY
#1150Target gene expression control system comprising dxCas9 and CRP derivative and preparation method therefor
#1151COMPOSITIONS AND METHODS FOR TREATMENT OF CANCERS USING MODIFIED siRNA-GEM AGENTS
#1152COMPOSITIONS AND METHODS FOR TREATING ALZHEIMER'S DISEASE UTILIZING A TRANSCRIPTIONAL MASTER REGULATOR OF THE RETROMER COMPLEX
#1153COMPOSITIONS FOR INHIBITING DIPEPTIDE REPEAT PROTEIN-RIBOSOMAL RNA INTERACTION AND USES THEREOF
#1154USE OF MIRNA-2911 MOLECULE AS NUCLEIC ACID STABILIZER
#1155STAGGERED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS
#1156METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION
#1157COMPLEMENT FACTOR B (CFB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1158USE OF FANA ANTISENSE OLIGONUCLEOTIDES FOR THE PREVENTION AND MANAGEMENT OF HUANGLONGBING AND ZEBRA CHIP DISEASES
#1159ENGINEERED NUCLEASES THAT TARGET HUMAN AND CANINE FACTOR VIII GENES AS A TREATMENT FOR HEMOPHILIA A
#1160Compositions And Methods For Differentiation Of Human Pluripotent Stem Cells Into Desired Cell Types
#1161MUSCLE TARGETING COMPLEXES FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#1162TISSUE-SPECIFIC IMAGING AND THERAPEUTIC AGENTS TARGETING PROTEINS EXPRESSED ON MUSCLE CELL SURFACE
#1163MESENCHYMAL STROMAL CELL DELIVERY VIA CARDIOPULMONARY BYPASS PROVIDES NEUROPROTECTION
#1164THERAPEUTIC NUCLEIC ACIDS AND METHODS OF USE THEREOF
#1165ANTICANCER COMPOSITIONS AND METHODS FOR MAKING AND USING THEM
#1166HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS
#1167Deaminase-Based RNA Sensors
#1168PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING TARGET CANCER INCLUDING BRCA-SPECIFIC siRNA AS ACTIVE INGREDIENT
#1169ANTITUMORAL COMPOSITION
#1170PHARMACEUTICAL COMPOSITION FOR PREVENTION OR TREATMENT OF BLOOD CANCER COMPRISING SURF4 INHIBITOR
#1171GATA4-TARGETED THERAPEUTICS FOR TREATMENT OF CARDIAC HYPERTROPHY
#1172TREATMENT FOR INFLAMMATORY DISEASE
#1173TREATING CHEMORESISTANT FORMS OF LEUKEMIA AND OTHER CANCERS THAT OVEREXPRESS RNA BINDING PROTEIN FXR1
#1174COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#1175IRNA COMPOSITIONS AND METHODS FOR SILENCING COMPLEMENT COMPONENT 3 (C3)
#1176MODIFIED U6 PROMOTER SYSTEM FOR TISSUE SPECIFIC EXPRESSION
#1177USE OF GANODERMA FUNGAL RNA MOLECULES, DRUG, DRUG COMPOSITION AND DELIVERY CARRIER
#1178ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV)
#1179DOSING OF MUSCLE TARGETING COMPLEXES FOR TREATING DYSTROPHINOPATHIES
#1180LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY
#1181PHARMACEUTICAL COMPOSITION FOR PROMOTING CANCER IMMUNOTHERAPY AND METHOD FOR PROMOTING CANCER IMMUNOTHERAPY
#1182LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1183YEAST STRAIN FOR MOSQUITO MANAGEMENT
#1184Compositions and Methods for Modulating Single Stranded DNA Regions that Catalyze Enzymatic Reactions
#1185RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS
#1186GENE THERAPY FOR NEURODEGENERATIVE DISORDERS
#1187ARTIFICIAL YEAST PROMOTER REGIONS
#1188METHODS AND COMPOSITIONS TARGETING NUCLEUS ACCUMBENS-ASSOCIATED PROTEIN-1 FOR TREATMENT OF AUTOIMMUNE DISORDERS AND CANCERS
#1189COMPOSITIONS OF HUMAN HEART DERIVED EXTRACELLULAR VESICLES AND USES THEREOF
#1190COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS
#1191APP iRNA Compositions and Methods of Use Thereof for Treating or Preventing Diseases Characterized by Enlarged Endosomes
#1192DELIVERY OF ANITSENSE OLIGOMERS BY MIRROR IMAGE PEPTIDES
#1193HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1194Engineered Guide RNAs and Polynucleotides
#1195ANTISENSE COMPOUNDS AND METHODS FOR TARGETING CUG REPEATS
#1196COMPOSITIONS AND METHODS FOR TREATING TDP-43 PROTEINOPATHY
#1197NEURODEGENERATIVE DISORDERS
#1198METHODS OF EDITING WITH ENGINEERED CLASS 2 TYPE V CRISPR SYSTEMS
#1199TARGETING APOE ENHANCES T-CELL KILLING IN CANCER IMMUNOTHERAPY
#1200OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME