109054 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides against enzymes
INTERFERING RNA FOR INHIBITING JAK1 GENE EXPRESSION AND USE THEREOF
#2RNA-BASED COMPOSITIONS AND METHODS OF USE THEREOF
#3Nucleic acid regulation of c9orf72
#4COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#5DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE
#6MICROPARTICLE, PREVENTIVE DRUG OR THERAPEUTIC DRUG FOR ERECTILE DYSFUNCTION, AND METHOD FOR IMPROVING ERECTILE DYSFUNCTION
#7ANTISENSE OLIGONUCLEOTIDES FOR TREATING A DISEASE OR CONDITION ASSOCIATED WITH AN ABNORMAL PROCESSING OF APP
#8NOVEL MICROBIAL GENOTOXINS
#9Treatment Of Decreased Bone Mineral Density With Zinc And Ring Finger 3 (ZNRF3) Inhibitors
#10RNAi Agent Targeting PCSK9 and Use Thereof
#11INTERFERING RNA FOR INHIBITING TOP1 GENE EXPRESSION AND USE THEREOF
#12COMPOSITIONS AND METHODS FOR DELIVERING A MACROMOLECULE TO A CELL
#13RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use
#14GENE THERAPY FOR PRADER WILLI SYNDROME
#15COMPOSITION AND METHODS TO REDUCE INFLAMMATION AND PROMOTE REJUVENATION
#16METHODS OF TREATING CANCERS
#17THERAPEUTIC AGENT FOR TREATING HIF-1alpha-MEDIATED DISEASES BY INHIBITING AREL1 AND RESTORING PHD2 ACTIVITY
#18NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#19TREATMENT OF CANCERS HAVING A DRUG-RESISTANT MESENCHYMAL CELL STATE
#20CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT
#21USE OF TNKS INHIBITORS FOR REGENERATION OF CARTILAGE
#22PLATELETS TRANSFECTED WITH SIRNA AND THE THERAPEUTICS USES THEREOF
#23ANTISENSE OLIGONUCLEOTIDE, COMPOSITIONS AND PHARMACEUTICAL FORMULATIONS THEREOF FOR EXON SKIPPING
#24ANTIBACTERIAL PHAGE, THERAPEUTIC COMPOSITION, BACTERICIDAL AGENT, FOOD, BACTERIA IDENTIFICATION KIT, THERAPEUTIC COMPOSITION MANUFACTURING METHOD, BACTERIA ELIMINATION METHOD, BACTERIA IDENTIFICATION METHOD, AND ANIMAL THERAPEUTIC METHOD
#25METHODS OF TREATING MYELODYSPLASTIC SYNDROME
#26Compounds and Methods for Reducing ATXN3 Expression
#27COMPOSITIONS AND METHODS TO MODULATE TUMOR MICROENVIRONMENT ASSOCIATED LONG NONCODING RNAS
#28THERAPY BY TRANS-SPLICING OF OPA1 PRE-MESSENGER RNAS FOR THE TREATMENT OF DISEASES ASSOCIATED WITH OPA1 GENE MUTATIONS
#29Methods for Preventing Cardiovascular Events Through Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Reduction
#30ANTISENSE OLIGONUCLEOTIDES FOR THE TREATMENT OF CANAVAN DISEASE
#31MICROPARTICLE, AGENT FOR ACTIVATING NK CELL, METHOD FOR CULTURING NK CELL, METHOD FOR PRODUCING ACTIVATED NK CELL, AND METHOD FOR ACTIVATING NK CELL
#32ANTI-FIBROTIC MICRORNA COMPOSITION
#33PKC INHIBITORS FOR THE TREATMENT OF SEPTIC CHOLESTASIS WITH POLYMETHINE DYE TARGETING
#34COMPOSITIONS AND METHODS TO TREAT ALZHEIMER'S DISEASE AND OTHER BRAIN DISEASES
#35Treatment Of Respiratory Disorders With Arachidonate 15-Lipoxygenase (ALOX15) Inhibitors
#36NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#37IRON METABOLISM TARGETS FOR OBESITY
#38GALNAC MONOMER COMPRISING RIBOSE RING OR DERIVATIVE STRUCTURE THEREOF AND USE THEREOF IN LIVER-TARGETED DELIVERY OF SMALL NUCLEIC ACID DRUGS
#39COMPOSITIONS FOR USE IN THE TREATMENT OF CHD2 HAPLOINSUFFICIENCY
#40PLANTS GENETICALLY ENGINEERED FOR INCREASED WATER USE EFFICIENCY AND CARBON INTAKE AND METHODS FOR MAKING AND USING THEM
#41Use of a Janus Kinase Inhibitor and a Telomerase Inhibitor for the Treatment of Myeloproliferative Neoplasms
#42Treatment Of Sepsis With PCSK9 And LDLR Modulators
#43LIPOSOMAL NANOCARRIER DELIVERY SYSTEM FOR TARGETING ACTIVE CD44 MOLECULE, PREPARATION METHOD THEREFOR, AND USES THEREOF
#44COMPOSITIONS AND METHODS FOR THE DELIVERY OF ACTIVE AGENTS INCLUDING NUCLEIC ACIDS
#45Treatment Of Pan-Cancer Phenotype With Regulator of Telomere Elongation Helicase 1 (RTEL1) Inhibitors
#46TREATMENT FOR OVARIAN CANCER WITH OLIGONUCLEOTIDES TARGETING FIBROBLAST ACTIVATION PROTEIN ALPHA
#47COMPOSITIONS AND METHODS FOR INHIBITING XDH EXPRESSION
#48RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITING EXPRESSION OF DYSTROPHIA MYOTONICA PROTEIN KINASE AND/OR INTERFERING WITH A TRINUCLEOTIDE REPEAT EXPANSION IN THE 3' UNTRANSLATED REGION OF THE DMPK GENE
#49TREM2 BINDS TO SPECIFICALLY STRUCTURED HEPARAN SULFATE
#50INHIBITION OF PLANT PROTEASE AED3-1 FOR IMPROVED HETEROLOGOUS PROTEIN PRODUCTION
#51GalNAc Compound Containing Triazole Structure and Oligonucleotide Conjugate Thereof
#52ANTISENSE OLIGONUCLEOTIDE FOR INHIBITING ACSL4 GENE EXPRESSION AND ITS APPLICATIONS
#53SOD1 DUAL EXPRESSION VECTORS AND USES THEREOF
#54EXPRESSION OF FC-CONTAINING PROTEINS
#55MODIFIED IMMUNE CELLS AND USES THEREOF
#56METHODS OF ALTERING THE STARCH GRANULE PROFILE IN PLANTS
#57COMPOSITIONS AND METHODS FOR INHIBITING ADENYLATE CYCLASE 9 (AC9)
#58Oligonucleotide for reducing the expression of leucine-rich repeat kinase 2 (LRRK2) and its use for preventing and/or treating human diseases
#59METHODS FOR TREATING ENDOMETRIAL AND OVARIAN HYPERPROLIFERATIVE DISORDERS
#60PLASMINOGEN (PLG) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#61METHODS AND COMPOSITIONS FOR TARGETING SERINE DEHYDRATASE
#62COMPRISING EXOSOMAL MIR-664A-5P AS AN ACTIVE INGREDIENT, A DIAGNOSTIC BIOMARKER COMPOSITION FOR PARP INHIBITOR RESPONSE AND A PHARMACEUTICAL COMPOSITION FOR CANCER TREATMENT
#63SYSTEMS AND METHODS FOR TARGETING NAD-BASED PATHWAYS FOR TREATMENT OF CANCER
#64KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#65HYBRID OLIGONUCLEOTIDES
#66AGENTS FOR MODULATING EXPRESSION
#67METHOD FOR PREPARING ENHANCED CAR-T-CELLS BASED ON INTERFERING OR KNOCKING OUT HUMAN PCSK9 GENE AND APPLICATION THEREOF
#68ASPARAGINE SYNTHETASE INHIBITORS AND USES THEREOF
#69SUBPOPULATION-DIRECTED REMEDIATION OF DISEASE-ASSOCIATED GENE PRODUCTS
#70Compositions and Methods for Modulating Complement Factor B Expression
#71RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use
#72GENETIC MODULATORS OF KRAS PROTEIN EXPRESSION AND THEIR USES
#73DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE
#74FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#75COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY
#76RNAi Agents for Inhibiting Expression of Mitochondrial Amidoxime Reducing Component 1 (MARC1), Pharmaceutical Compositions Thereof, and Methods of Use
#77INHIBITORS OF EXPRESSION AND/OR FUNCTION
#78GALNAC COMPOUND CONTAINING RIBOSE RING OR ITS DERIVATIVE STRUCTURE AND OLIGONUCLEOTIDE CONJUGATE THEREOF
#79ADENO-ASSOCIATED VIRUS GENE THERAPY PRODUCTS AND METHODS
#80COMPOSITIONS AND METHODS FOR TREATING PANCREATIC CANCER
#81OLIGONUCLEOTIDES FOR MODULATING RTEL1 EXPRESSION
#82SIRNA TARGETING AND REGULATING PCSK9 GENE EXPRESSION AND USE THEREOF
#83TARGETING CREB-HEPARAN SULFATE-FGF PATHWAY FOR CANCER TREATMENT
#84OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#85IMMUNE EFFECTOR CELL THERAPIES WITH ENHANCED EFFICACY
#86SIRNA TARGETING RECQL1 HELICASE GENE
#87DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS FOR RNA INTERFERENCE AND METHODS RELATING THERETO
#88COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY
#89METHODS AND COMPOSITIONS FOR CELL-PROLIFERATION-RELATED DISORDERS
#90RNAi Agents for Inhibiting Expression of Proprotein Convertase Subtilisin Kexin 9 (PCSK9), Pharmaceutical Compositions Thereof, and Methods of Use
#91COMBINATION VECTORS AND METHODS FOR TREATING CANCER
#92COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#93NUCLEOTIDE ANALOGUES, AND PREPARATION AND APPLICATION THEREOF
#94Compositions and Methods for GYS1 Inhibition
#95Targeted Nanomedicine for Treating Fibrotic Lung Disorders
#96MUSCLE TARGETING COMPLEXES AND FORMULATIONS FOR TREATING MYOTONIC DYSTROPHY
#97Inducing Proliferation of Cardiomyocytes and Therapeutic Uses Related Thereto
#98SYSTEMS FOR CELL PROGRAMMING AND METHODS THEREOF
#99PHARMACEUTICAL COMPOUND FOR PREVENTION OR TREATMENT OF LIVER FIBROSIS
#100INHIBITORY AGENT FOR MYOCARDIAL CELL DEATH, AND PROPHYLACTIC OR THERAPEUTIC AGENT FOR MYOCARDIAL DISORDERS OR HEART FAILURE
#101METHOD FOR TREATMENT OF MYOTONIC DYSTROPHY COMBINING PROTEIN EXPRESSION AND RNA INTERFERENCE VECTOR DELIVERY WITH TISSUE DETARGETING
#102USE OF CONJUGATES OF MICRORNA AND CARDIAC TARGETING PEPTIDES FOR TREATING HEART FAILURE
#103RNAI AGENT INHIBITING PCSK9 GENE EXPRESSION AND APPLICATION THEREOF
#104INTRACELLULAR KINASE ASSOCIATED WITH RESISTANCE AGAINST ANTI-TUMOUR IMMUNE RESPONSES, AND USES THEREOF
#105COMPOSITIONS AND METHODS FOR MODULATING CONDITIONS ASSOCIATED WITH ALTERED ATP8B1 FUNCTION
#106ANTISENSE OLIGOMERS AGAINST MONOAMINE OXIDASE B AND USE THEREOF
#107Method For Treating Cyclophilin B Associated Diseases
#108GLIOBLASTOMA TUMOR GROWTH INHIBITON BY SAT1 KNOCKDOWN
#109COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#110COMPOSITIONS AND METHODS FOR TREATING METABOLIC DYSFUNCTION-ASSOCIATED STEATOTIC LIVER DISEASE
#111Conjugated Antisense Compounds and Their Use
#112OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#11317ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#114INHIBITION OF HISTONE METHYL TRANSFERASES TO TREAT CANCER
#115METHOD FOR TESTING PULMONARY HYPERTENSION, PATHOLOGICAL ANIMAL MODEL FOR PULMONARY ARTERIAL HYPERTENSION, AND PREVENTIVE OR THERAPEUTIC AGENT FOR PULMONARY HYPERTENSION
#116METHOD FOR CARDIAC REPAIR
#117AAV VECTORS ENCODING SOD1-TARGETING ARTIFICIAL MIRNAS (AMI-RNA)
#118RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#119PALMITOYLATION OF THE ALTERNATIVE AMINO TERMINUS OF THE BTK-C ISOFORM CONTROLS SUBCELLULAR DISTRIBUTION AND SIGNALING
#120NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND SIRNA CONJUGATE CONTAINING THE NUCLEIC ACID, PREPARATION METHOD THEREFOR, AND USE THEREOF
#121NUCLEIC ACID MOLECULE FOR REDUCTION OF PAPD5 AND PAPD7 mRNA FOR TREATING HEPATITIS B INFECTION
#122IMPROVED PROTEIN PRODUCTION USING miRNA TECHNOLOGY
#123Compositions and Methods for Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Editing
#124INTERFERING RNA FOR INHIBITING PCSK9 GENE EXPRESSION AND USE THEREOF
#125METHODS FOR TREATING HYPERCHOLESTEROLEMIA
#126Compounds and Methods for Reducing LRRK2 Expression
#127PHARMACEUTICAL COMPOSITION FOR TREATING OR PREVENTING MALIGNANT BREAST CANCER
#128INHIBITORS OF EXPRESSION AND/OR FUNCTION
#129UBE3A ANTISENSE THERAPEUTICS
#13017BETA-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#131TREATMENT OF CARDIOVASCULAR DISEASE
#132HUMAN ANTIBODIES TO THE GLUCAGON RECEPTOR
#133METHOD OF SYNTHESIS OF AN IONIZABLE CATIONIC LIPID
#134SMALL RNA DRUG FOR INHIBITING ACTIVITY OF CANCER CELLS
#135SMALL RNA AND USE THEREOF IN TREATMENT OF HYPERLIPIDEMIA
#136OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#137COMPOSITIONS AND METHODS FOR INHIBITING CYTOCHROME P450 FAMILY 7 SUBFAMILY A MEMBER 1 (CYP7A1) EXPRESSION
#138ENGINEERED IMMUNE CELL WITH CIITA GENE KNOCK-OUT AND USE THEREOF
#139OLIGONUCLEOTIDE-BASED DELIVERY VEHICLE FOR OLIGONUCLEOTIDES AGENTS AND METHODS OF USE THEREOF
#140MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#141COMPOSITIONS AND METHODS OF MODULATING XANTHINE DEHYDROGENASE
#142MIRNA COMBINATION FOR THE PREVENTION AND TREATMENT OF CANCER
#143METHODS AND COMPOSITIONS FOR INHIBITING EXPRESSION OF LDHA
#144MODULATORS OF DIACYGLYCEROL ACYLTRANSFERASE 2 (DGAT2)
#145TREATMENT OF A NON-ALCOHOLIC FATTY LIVER DISEASE
#146TREATMENT OF CARDIOVASCULAR DISEASE
#147COMPOSITIONS FOR TREATING AND/OR PREVENTING CELL OR TISSUE NECROSIS SPECIFICALLY TARGETING CATHEPSIN C AND/OR CELA1 AND/OR CELA3A AND/OR STRUCTURALLY RELATED ENZYMES THERETO
#148POLYNUCLEOTIDE FOR TREATMENT OF NEURODEGENERATIVE DISEASE, VECTOR, CELL, PHARMACEUTICAL COMPOSITION, AND SCREENING METHOD
#149FN3 DOMAIN-siRNA CONJUGATES AND USES THEREOF
#150COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#151COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#152METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER
#153METHODS AND COMPOSITIONS FOR TREATING INFLAMMATORY CONDITIONS ASSOCIATED WITH INFECTIOUS DISEASE
#154CO-DELIVERY OF INHIBITORY NUCLEIC ACIDS AND GENOME EDITORS FOR TUMOR THERAPY
#155TARGETED AUGMENTATION OF NUCLEAR GENE OUTPUT
#156BIS-RNAI COMPOUNDS FOR CNS DELIVERY
#157FUNCTIONAL NUCLEIC ACID MOLECULES
#158LIPID NANOPARTICLES COMPRISING MANNOSE OR USES THEREOF
#159COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#160COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#161COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#162COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#163COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#164COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#165COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#166COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#167KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#168TREATMENT OF H3.3-MUTANT BRAIN CANCER WITH PNKP INHIBITORS
#169NON-HALLUCINOGENIC PSYCHEDELIC FUNGI
#170MODULATION OF GENE TRANSCRIPTION USING ANTISENSE OLIGONUCLEOTIDES TARGETING REGULATORY RNAS
#171SIRNA OR SALT THEREOF AND MEDICAMENT FOR INHIBITING EXPRESSION OF TMPRSS6 GENE, AND USE THEREOF
#172POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF FXI, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#173XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#174SARM1 RNAi AGENTS
#175DOSING OF MUSCLE TARGETING COMPLEXES FOR TREATING MYOTONIC DYSTROPHY
#176piRNA-BASED CONSTRUCTS FOR REGULATING GENE EXPRESSION AND METHODS OF USE THEREOF
#177COMPOSITIONS AND METHODS FOR PRODUCING TOBACCO PLANTS AND PRODUCTS HAVING ALTERED ALKALOID LEVELS WITH DESIRABLE LEAF QUALITY VIA MANIPULATING LEAF QUALITY GENES
#178PNPLA3-TARGETING SHORT INTERFERING RNA (SIRNA) MOLECULES AND USES THEREOF
#179Oligonucleotides
#180MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MYOTONIC DYSTROPHY
#181METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
#182Methods and Compositions for Inhibiting the Growth and/or proliferation of MYC-Driven Tumor Cells
#183RNA MOLECULES FOR TREATING FUNGI
#184Nucleic acids for inhibiting expression of MASP-2 in a cell
#185COMPOSITIONS AND METHODS FOR TREATMENT OF SEPSIS-RELATED DISORDERS
#186COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING GPAM
#187Process to Inhibit or Eliminate Eosinophilic Diseases of the Airway and Related Conditions
#188METHODS OF TREATING, AMELIORATING AND/OR PREVENTING FIBRODYSPLASIA OSSIFICANS PROGRESSIVA AND HETEROTOPIC OSSIFICATION, AND KITS FOR THE SAME
#189COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#190LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO CNS TISSUE
#191ANTISENSE NUCLEIC ACID CAPABLE OF INHIBITING BIOSYNTHESIS OF CHONDROITIN SULFATE
#192ANTI-HELICASE THERAPY FOR TREATMENT OF REPEAT EXPANSION DISEASE
#193COMPOSITION FOR PREVENTION OR TREATMENT OF CANCER COMPRISING DDX54 INHIBITOR AND CANCER IMMUNOTHERAPY AGENT
#194RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use
#195BICYCLIC HETEROCYCLES AND THEIR LIGANDS FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#196NOVEL APPROACH FOR TREATMENT OF CANCER USING IMMUNOMODULATION
#197RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use
#198RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#199Treatment Of Liver Disease With Mitochondrial Glycerol-3-Phosphate Acyltransferase (GPAM) Inhibitors
#200PHARMACEUTICAL COMPOSITION FOR TREATMENT OR PREVENTION OF FIBROTIC DISEASE
#201GENE EXPRESSION REGULATOR, AGENT FOR PREVENTING OR TREATING ALZHEIMER'S DISEASE AND METHOD FOR IMPROVING DEMENTIA
#202METHODS OF TREATING CHOLANGIOCARCINOMA
#203COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY
#204METHODS OF DESIGNING CONDITIONAL-ACTIVATABLE SMALL INTERFERING RNA SENSORS
#205KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#206TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS
#207Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors
#208SARM1 RNA INTERFERENCE AGENTS
#209NONCOVALENTLY BRANCHED OLIGONUCLEOTIDE COMPOSITIONS
#210MULTIPLEXING TARGETING LIGANDS THROUGH CLICK CHEMISTRY AT THE ANOMERIC SITE OF SUGARS
#211MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#212PYK2 INHIBITION MODULATES IMMUNE CELL FUNCTION
#213METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER TREATMENT BY INCREASING TUMOR MUTATION BURDEN OR TUMOR INDELS
#214PHARMACEUTICAL COMPOSITION COMPRISING SETMAR INHIBITOR FOR PREVENTING OR TREATING CANCER
#215USE OF CDK16 AS TARGET IN PREPARATION OF MEDICINE FOR TREATING TRIPLE-NEGATIVE BREAST CANCER
#216RNAI AGENT TARGETING MARC1 GENE, AND USE THEREOF
#217COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#218APPLICATION OF MECHANICAL-FORCE SENSITIVE MACROPHAGE SUBSET IN PANCREATIC CANCER DIAGNOSIS OR PROGNOSIS EVALUATION
#219ANTISENSE-INDUCED EXON2 INCLUSION IN ACID ALPHA-GLUCOSIDASE
#220ANTISENSE OLIGOMERS AND METHODS OF USING THE SAME FOR TREATING DISEASES ASSOCIATED WITH THE ACID ALPHA-GLUCOSIDASE GENE
#221GENE THERAPEUTICS FOR TREATING BONE DISORDERS
#222MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#223COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#224COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#225COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#226COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#227COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#228COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#229COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#230COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#231COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#232BRAIN TUMOR MODEL
#233RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#234Products and Methods for Treatment of Amyotrophic Lateral Sclerosis
#235COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#236COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PREKALLIKREIN (PKK) PROTEIN
#237Transdifferentiation of Pancreatic Duct Cells Into Beta-Like Cells
#238COMPOSITIONS AND METHODS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN HUMAN ANGELMAN SYNDROME
#239TREATMENT FOR SOD1 ASSOCIATED DISEASE
#240ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF
#241METHOD OF MAKING BONE AND CARTILAGE
#242ANTISENSE OLIGONUCLEOTIDES TARGETING ADENOSINE KINASE
#243NUCLEIC ACID MODIFIED BIOLOGICAL CELL WITH EXPANSION-DEPENDENT GENE EXPRESSION
#244Treatment Of Osteoarthritis With Procollagen Galactosyl Transferase 2 (COLGALT2) Inhibitors
#245Treatment Of Macular Degeneration With Complement Factor D (CFD) Inhibitors
#246METHOD FOR REDUCING HEPATIC TRIGLYCERIDES
#247COMPOSITIONS AND METHODS FOR TREATING CORONAVIRUS INFECTIOUS DISEASE-19 (COVID-19)
#248COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#249COMBINATIONS WITH MODULATORS OF PNPLA3 EXPRESSION
#250IMMUNE CELLS WITH ENHANCED EFFICACY
#251OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#252Treatment Of Uveitis With Endoplasmic Reticulum Aminopeptidase 1 (ERAP1) Inhibitors
#253MODULATORY POLYNUCLEOTIDES
#254MODULATION OF SUV39H1 EXPRESSION BY RNAS
#255PREKALLIKREIN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#256COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA
#257COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEASES AND NEUROGENERATIVE DISORDERS
#258COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS
#259DEGRADATION OF RNA BY THE LYSOSOMAL PATHWAY
#260ANTISENSE OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTION OR TREATMENT OF GLYCOGEN STORAGE DISEASE TYPE IA
#261PIKFYVE ANTISENSE OLIGONUCLEOTIDES
#262COMPOSITIONS AND METHODS FOR INHIBITING KETOHEXOKINASE (KHK)
#263Treatment Of Acne Rosacea With Pancreatic Lipase-Related Protein 3 (PNLIPRP3) Inhibitors
#264COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#265HEPARIN SULFATE BIOSYNTHESIS PATHWAY ENZYME IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#266TARGETING OF XKR8 IN THERAPIES
#267PHARMACEUTICAL COMPOSITION FOR SUPPRESSING INVASION OF CANCER, AND METHOD FOR SUPPRESSING INVASION OF CANCER
#268COMPOSITIONS AND METHODS FOR TREATING CANCER
#269m6A mRNA MODIFICATION IN CANCER TREATMENT
#270PREKALLIKREIN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#271MEANS AND METHOD FOR PREPARING VIRAL VECTORS AND USES OF SAME
#272Application of PRDX5 and GPX4 Genes in Preparation of Drugs for Castration-resistant Prostate Cancer
#273ANTI-SENSE OLIGONUCLEOTIDES AND USES THEREOF
#274COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEIN KINASE (DMPK) EXPRESSION
#275RNA INTERFERENCE MEDIATED INHIBITION OF PROLYL HYDROXYLASE DOMAIN 2 (PHD2) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#276COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#277METHODS FOR THE TREATMENT OF NLRP3 RELATED DISORDERS
#278ENHANCED PRODUCTION OF SQUALENE IN PLANT SYSTEMS
#279Guide RNA That Targets A Mutant Human Guanylate Cyclase 2A Allele
#280Exosomes for treating glioblastoma multiforme and manufacturing method thereof
#281METHODS AND COMPOSITIONS RELATED TO RNA-TARGETED RHO SMALL GTPase RND3/RhoE THERAPY
#282COMPOUNDS AND METHODS FOR MODULATING GLYCOGEN SYNTHASE 1
#283COMPOSITIONS AND METHODS FOR MODULATING mRNA SPLICING
#284FERROCHELATASE INHIBITORS AND METHODS OF USE
#2853-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#286RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Compositions Thereof, and Methods of Use
#287Double Stranded Oligonucleotide For Modulating JAK1 Expression
#288OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS
#289METHODS OF SILENCING EXPRESSION OF GENES AND USES THEREOF
#290COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#291COMPOSITIONS AND METHODS FOR TREATING FAN1 ASSOCIATED TRINUCLEOTIDE REPEAT EXPANSION DISORDERS
#292Compositions and Methods of Generating Novel amiRNA
#293MODULATING EXPRESSION OF ALAS1 (5'-AMINOLEVULINATE SYNTHASE 1) GENE
#294USE OF FANA ANTISENSE OLIGONUCLEOTIDES FOR THE PREVENTION AND MANAGEMENT OF HUANGLONGBING AND ZEBRA CHIP DISEASES
#295NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF TMPRSS6 AND IRON CHELATORS
#296METHODS OF TARGETING RNF213 SIGNALING PATHWAY FOR TREATING DISEASES
#297NOVEL OXO-RNA COMPOSITIONS AND THE RELATED APPLICATIONS THEREOF
#298METHODS FOR THE TREATMENT OF HRD CANCER AND BRCA-ASSOCIATED CANCER
#299AGENTS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS
#300Methods for the Modification of Cells, Modified Cells and Uses Thereof