109132 ⎘
Structure or type of the nucleic acid; Type of nucleic acid Antisense
COMPOUNDS FOR TREATMENT OF CONDITIONS AND DISEASES
#302OVERSUBSCRIPTION SCHEDULING
#303COMPOSITIONS AND METHODS FOR INHIBITING STAG1 EXPRESSION AND USES THEREOF
#304MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MYOTONIC DYSTROPHY
#305POLY-GA PROTEINS IN ALZHEIMER’S DISEASE
#306Methods Of Treating Decreased Bone Mineral Density With Cluster Of Differentiation 109 (CD109) Inhibitors
#307EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#308RNA MOLECULES FOR TREATING FUNGI
#309Novel systems for nucleic acid regulation
#310METHODS OF TREATMENT OF GNAQ AND GNA11 DRIVEN DISEASE
#311CARBOCYCLIC NUCLEOSIDE, OLIGONUCLEOTIDE AND PREPARATION METHODS THEREFOR AND MEDICAL USES THEREOF
#312INTRACELLULAR TARGETING OF OLIGONUCLEOTIDES
#313Process to Inhibit or Eliminate Eosinophilic Diseases of the Airway and Related Conditions
#314COMBINATION OF A GREMLIN-1 ANTAGONIST WITH AN INHIBITOR OF RAS-RAF-MEK-ERK SIGNALLING
#315COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#316CHEMICALLY MODIFIED SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
#317SYF2 ANTISENSE OLIGONUCLEOTIDES
#318Selective Reduction of Allelic Variants
#319OLIGONUCLEOTIDES WITH 2'-DEOXY-2'-F-2'-C-METHYL NUCLEOTIDES
#320TRANS-VACCENIC ACID (TVA) AND DERIVATIVES THEREOF IN T CELL-BASED CANCER THERAPIES
#321Antisense Nucleic Acids for Use in the Treatment for KCNQ1 Mutation Carriers
#322METHOD OF TREATING CHRONIC HEPATITIS B
#323MODULATION OF HEPATITIS B VIRUS (HBV) EXPRESSION
#324COMPOSITIONS AND METHODS FOR THE TREATMENT OF MUSCULAR DYSTROPHIES
#325COMPOSITIONS AND METHODS FOR RECOMBINANT AAV PRODUCTION
#326TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE
#327METHODS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#328POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF
#329PHYTOECDYSONES AND/OR 20-HYDROXYECDYSONE DERIVATIVES IN COMBINATION WITH AN ACTIVE INGREDIENT FOR RESTORING SMN EXPRESSION, FOR USE IN THE TREATMENT OF SPINAL MUSCULAR ATROPHY
#330THERAPEUTIC VESICLES AND METHODS OF PROCESSING THE SAME
#331Viral Vectors For Treating Neurogenic Detrusor Overactivity
#332PHARMACEUTICAL COMPOSITION FOR TREATMENT OR PREVENTION OF FIBROTIC DISEASE
#333COMPOSITIONS AND USES FOR TREATMENT THEREOF
#334COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES
#335RNAi Agents of Modulating PLP1
#336METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#337COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE
#338SIRNA TARGETING ANGIOTENSINOGEN AND PHARMACEUTICAL USE OF SIRNA
#339METHODS OF TREATING CHOLANGIOCARCINOMA
#340siRNA SUPPRESSING EXPRESSION OF TRANSFERRIN RECEPTOR 2
#341COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION
#342TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS
#343Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors
#344SARM1 RNA INTERFERENCE AGENTS
#345MULTIPLEXING TARGETING LIGANDS THROUGH CLICK CHEMISTRY AT THE ANOMERIC SITE OF SUGARS
#346ANTIVIRAL ANTISENSE OLIGOMER
#347POLYNUCLEIC ACID MOLECULES TARGETING APOC3 AND USES THEREOF
#348POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF LP(A), PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#349ANTISENSE OLIGONUCLEOTIDES FOR TARGETING PROGRANULIN
#350METHODS OF TREATING OSMIDROSIS
#351CHIMERIC RNA-DRIVEN GENOMIC REARRANGEMENT IN MAMMALIAN CELLS
#352Antisense Nucleic Acids
#353COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLIOBLASTOMA BY INHIBITION OF THE TFPI2-CD51-STAT6 SIGNALING AXIS
#354METHOD FOR TREATING CLONAL HEMATOPOIETIC BLOOD DISORDERS
#355MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#356METHODS OF USING OLIGOMERIC COMPOUNDS TO TREAT SCN2A-RELATED DISORDERS
#357METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER TREATMENT BY INCREASING TUMOR MUTATION BURDEN OR TUMOR INDELS
#358RNAI AGENT TARGETING MARC1 GENE, AND USE THEREOF
#359ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#360COMPOUNDS AND METHODS FOR MODULATING SMN2
#361METHODS OF TREATING GLAUCOMA
#362EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#363HETERONUCLEIC ACID INCLUDING 2'-MODIFIED NUCLEOSIDE
#364MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#365CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE
#366G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC
#367TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIOID ANALGESICS
#368ANTISENSE-INDUCED EXON2 INCLUSION IN ACID ALPHA-GLUCOSIDASE
#369COMPOSITIONS, SYSTEMS, AND METHODS FOR REGULATION OF HEPATITIS B VIRUS THROUGH TARGETED GENE REPRESSION
#370Linear DNA with Enhanced Resistance Against Exonucleases
#371ANTISENSE OLIGOMERS AND METHODS OF USING THE SAME FOR TREATING DISEASES ASSOCIATED WITH THE ACID ALPHA-GLUCOSIDASE GENE
#372NON-CANONICAL CELL-PENETRATING PEPTIDES FOR ANTISENSE OLIGOMER DELIVERY
#373MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#374NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON SKIPPING
#375INHIBIN SUBUNIT BETA E INHIBITOR AND METHODS OF USE THEREOF
#376METHODS FOR IMMUNOREGULATION BY MODULATING PLASMINOGEN-APPLE-NEMATODE (PAN) DOMAIN-CONTAINING PROTEINS
#377INTRON FRAGMENTS
#378Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#379THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS
#380ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF
#381TRIMERIC PEPTIDES FOR ANTISENSE DELIVERY
#382COMPOUND FOR INHIBITING C3 GENE EXPRESSION, PHARMACEUTICAL COMPOSITION AND USE THEREOF
#383NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON SKIPPING
#384MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
#385MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#386Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#387Compositions and Methods for Enhancing AAV Therapy and Decreasing Tropism of AAV to the Liver
#388Antisense Nucleic Acids
#389OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES
#390ENHANCED EXPRESSION OF ALTERNATIVE SPLICED UROMODULIN FOR THERAPEUTICUSE
#391EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#392TRANS-SPLICING RNA (TSRNA)
#393Ventricular Arrhythmias and Related Methods
#394TREATMENT OF SMOKING WITH CHOLINERGIC RECEPTOR NICOTINIC BETA 3 SUBUNIT (CHRNB3) INHIBITORS
#395SPLICE-SWITCHING OLIGONUCLEOTIDES AND METHODS OF USE
#396TREATMENT FOR SOD1 ASSOCIATED DISEASE
#397ANTISENSE OLIGONUCLEOTIDES TARGETING ADENOSINE KINASE
#398COMPOSITIONS, SYSTEMS, AND METHODS FOR REGULATION OF HEPATITIS B VIRUS THROUGH TARGETED GENE REPRESSION
#399ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF
#400CHANNEL MODULATORS
#401MODULATORS OF MALAT1 EXPRESSION
#402OLIGONUCLEOTIDE AGONISTS TARGETING PROGRANULIN
#403MODULATION OF ALPHA SYNUCLEIN EXPRESSION
#404METHODS TO ACCELERATE STEM CELL DIFFERENTIATION TO CARDIOMYOCYTES
#405CELL-PENETRATING PEPTIDES FOR ANTISENSE DELIVERY
#406Targeting Oncogenic KRAS with Molecular Brush-Conjugated Antisense Oligonucleotide
#407Treatment Of Myeloid Cell Dysfunction With Membrane Spanning 4-Domains A6A (MS4A6A) Inhibitors
#408METHODS AND SYSTEMS FOR INDUCING APOPTOSIS OF ADIPOSE CELLS
#409Treatment Of Osteoarthritis With Procollagen Galactosyl Transferase 2 (COLGALT2) Inhibitors
#410Treatment Of Macular Degeneration With Complement Factor D (CFD) Inhibitors
#411METHOD FOR REDUCING HEPATIC TRIGLYCERIDES
#412COMPOSITIONS, SYSTEMS, AND METHODS FOR REGULATION OF HEPATITIS B VIRUS THROUGH TARGETED GENE REPRESSION
#413siRNA based on RNA sequence of SARS-CoV-2 and use thereof
#414CD71 BINDING FIBRONECTIN TYPE III DOMAINS
#415ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF
#416Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription
#417Therapeutic Compounds for Red Blood Cell-Mediated Delivery of an Active Pharmaceutical Ingredient to a Target Cell
#418COMBINATIONS WITH MODULATORS OF PNPLA3 EXPRESSION
#419Bifunctional Molecules and Methods of Using Thereof
#420RNAi OLIGONUCLEOTIDE CONJUGATES
#421ARTIFICIAL NUCLEIC ACIDS FOR RNA EDITING
#422COMPOSITIONS OF LEUKOCYTES WITH RESISTANCE TO PROSTANOIDS AND RELATED METHODS OF USE
#423OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#424Treatment Of Uveitis With Endoplasmic Reticulum Aminopeptidase 1 (ERAP1) Inhibitors
#425PREKALLIKREIN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#426COMPOUNDS FOR INHIBITION OF IL-1BETA EXPRESSION
#427METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS
#428SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE
#429MODULATING THE CELLULAR STRESS RESPONSE
#430METHOD OF INTERFERING WITH REPETITIVE RNA
#431EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
#432LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF
#433THERAPY FOR POLYCYSTIC KIDNEY DISEASE
#434PRE-MRNA SLICE MODULATING PEPTIDE-CONJUGATED ANTISENSE THERAPEUTICS FOR THE TREATMENT OF DISEASES
#435COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEASES AND NEUROGENERATIVE DISORDERS
#436RIG1 Inhibition and Therapeutic Viral Protein Expression
#437COMPOUNDS AND METHODS FOR MODULATING PROGRANULIN EXPRESSION
#438COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS
#439TRIGGER NUCLEIC ACIDS AND RNA-BINDING PROTEINS FOR UPREGULATING GENE EXPRESSION
#440COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#441METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS
#442DEGRADATION OF RNA BY THE LYSOSOMAL PATHWAY
#443ANTISENSE OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTION OR TREATMENT OF GLYCOGEN STORAGE DISEASE TYPE IA
#444siRNAs and shRNAs Targeting HIV and Combinations, Expression Cassettes, Cells and Use Thereof
#445COMPOSITIONS AND METHODS FOR USING PURIFIED HUMAN RNA EDITING ENZYMES
#446OLIGONUCLEOTIDE MODULATORS ACTIVATING UTROPHIN EXPRESSION
#447MODIFIED siRNA FOR SELECTIVELY INHIBITING EXPRESSION OF MUTANT FUS
#448ALLELE SPECIFIC SPLICE SWITCHING OLIGONUCLEOTIDES TARGETING PSEUDOEXONS
#449CHEMICALLY MODIFIED ANTISENSE OLIGONUCLEOTIDES (ASOS) AND COMPOSITIONS COMPRISING THE SAME FOR RNA EDITING
#450Implantable Medical Device for the Delivery of a Nucleic Acid
#451MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA
#452PIKFYVE ANTISENSE OLIGONUCLEOTIDES
#453COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTIONS
#454Modified Oligonucleotides and Methods of Use
#455Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors
#456A GLUN2D INHIBITOR FOR USE IN THE TREATMENT OR RELAPSE PREVENTION OF A DEPRESSIVE EPISODE
#457EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#458ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATMENT OF NEURODEGENERATIVE DISORDERS
#459TREATMENT AND PREVENTION OF ALCOHOLIC LIVER DISEASE
#460EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#461COMPOSITIONS AND METHODS FOR TREATING CMT1A OR CMT1E DISEASES WITH RNAI MOLECULES TARGETING PMP22
#462Treatment Of Acne Rosacea With Pancreatic Lipase-Related Protein 3 (PNLIPRP3) Inhibitors
#463METHODS AND COMPOSITIONS TO REGULATE MAPT SPLICING FOR MODELING AND TREATMENT OF TAUOPATHIES
#464Antisense Nucleic Acids
#465Antisense Nucleic Acid
#466METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS
#467LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS
#468LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS
#469COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND TARGETED SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS
#470HIF1A OR GLUT1 INHIBITION IN INFLAMMATORY SKIN DISEASES
#471PEPTIDE LIGANDS FOR CNS AND OCULAR DELIVERY OF RNAI COMPOUNDS
#472Treatment Of Muscle Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors
#473L-RNA APTAMERS, RECOMBINANT POLYNUCLEOTIDES, AND USES THEREOF IN TREATING ALZHEIMERS DISEASE
#474RNAS FOR COMPLEMENT INHIBITION
#475METHODS AND COMPOSITIONS FOR TREATING PANCREATIC DISEASE
#476AGENTS AND METHODS FOR PREVENTING OR INHIBITING ADAPTIVE IMMUNE RESPONSES ASSOCIATED WITH MULTIPLE SCLEROSIS
#477DOUBLE-STRANDED RNA HAVING NUCLEOTIDE ANALOG
#478DETECTION OF GENETIC VARIANTS OF THE BETA-ADRENERGIC RECEPTOR PATHWAY FOR DETECTING AND TREATING RETINOPATHY OF PREMATURITY
#479ACVR1R206H ALLELE-SPECIFIC THERAPY AND USES THEREOF FOR TREATMENT OF FIBRODYSPLASIA OSSIFICANS PROGRESSIVA
#480ANTI-SENSE OLIGONUCLEOTIDES AND USES THEREOF
#481COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEIN KINASE (DMPK) EXPRESSION
#482ANTISENSE OLIGONUCLEOTIDES FOR MODIFYING PROTEIN EXPRESSION
#483MODULATORS OF APOL1 EXPRESSION
#484Novel Retinitis Pigmentosa Treatment
#485METHODS FOR TREATING CONDITIONS AND DISEASES
#486OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING
#487Advanced RNA targeting (ARNATAR) for angiotensinogen
#488METHODS AND AGENTS FOR INCREASING RBM3 EXPRESSION
#489ANTISENSE OLIGOMERS FOR TREATMENT OF CHRONIC KIDNEY DISEASE
#490OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#491AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENTS
#492MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF
#493DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF
#494IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#495COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH
#496NLRP3 oligonucleotide for use in preventing and/or treating an inflammatory disease
#497METHODS FOR TREATING BLADDER CANCER
#498ANTISENSE OLIGONUCLEOTIDES (ASOS) THAT SUPPRESS SARS-COV-2 REPLICATION
#499SNCA-TARGETING SIRNA COMPOSITIONS FOR TREATING SNCA-ASSOCIATED DISEASE
#500DOUBLE STRANDED RNA TARGETING ANGIOPOIETIN-LIKE 3 (ANGPTL-3) AND METHODS OF USE THEREOF
#501SGLT-2 TARGETING OLIGONUCLEOTIDES
#502THERAPEUTIC OLIGONUCLEOTIDES HAVING AN INTER-NUCLEOSIDE AMIDE LINKAGE
#503TUNABLE REVERSIR TM COMPOUNDS
#504ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDITING WITH ENDOGENOUS ADENOSINE DEAMINASE ACTING ON RNA (ADAR)
#505METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS
#506COMPOSITIONS AND METHODS FOR MODULATING mRNA SPLICING
#507INHIBIN SUBUNIT BETA E (INHBE) MODULATOR COMPOSITIONS AND METHODS OF USE THEREOF
#508OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#509OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
#510THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#511Antisense Oligonucleotide for Targeting Progranulin
#512COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS
#513ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA
#514TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE TRANSCRIPTS
#515COMPOSITIONS AND METHODS FOR MODULATING INTERFERON REGULATORY FACTOR-5 (IRF-5) ACTIVITY
#516Antisense Compounds Targeting Genes Associated with Cystic Fibrosis
#517FERROCHELATASE INHIBITORS AND METHODS OF USE
#518METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#519OLIGONUCLEOTIDES FOR SNCA MODULATION
#520PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS VIA FAST-FLOW SYNTHESIS
#521TREATMENT OF FGG RELATED DISEASES AND DISORDERS
#522ANTISENSE NUCLEIC ACIDS
#523OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS
#524METHODS OF SILENCING EXPRESSION OF GENES AND USES THEREOF
#525ANTISENSE OLIGONUCLEOTIDE DRUG TARGETS
#526Methods and Compositions for ADAR-Mediated Editing
#527Methods and Compositions for ADAR-Mediated Editing
#528Novel Compositions for Conjugating Oligonucleotides and Carbohydrates
#529COMPOSITIONS AND METHODS FOR TREATING FAN1 ASSOCIATED TRINUCLEOTIDE REPEAT EXPANSION DISORDERS
#530TARGETED VESICLE COMPOSITIONS AND METHODS
#531METHODS FOR CREATING BILAYERS FOR USE WITH NANOPORE SENSORS
#532DOUBLE STRANDED RNA TARGETING PROPROTEIN CONVERTASE SUBTILISIN KEXIN 9 (PCSK9) AND METHODS OF USE THEREOF
#533STAGGERED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS
#534METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION
#535COMPLEMENT FACTOR B (CFB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#536USE OF FANA ANTISENSE OLIGONUCLEOTIDES FOR THE PREVENTION AND MANAGEMENT OF HUANGLONGBING AND ZEBRA CHIP DISEASES
#537TISSUE-SPECIFIC IMAGING AND THERAPEUTIC AGENTS TARGETING PROTEINS EXPRESSED ON MUSCLE CELL SURFACE
#538ANTISENSE OLIGONUCLEOTIDE FOR REGULATING BCL2L12 EXPRESSION AND THE USE THEREOF IN TREATMENT OF DISEASES
#539GATA4-TARGETED THERAPEUTICS FOR TREATMENT OF CARDIAC HYPERTROPHY
#540TREATMENT FOR INFLAMMATORY DISEASE
#541TREATING CHEMORESISTANT FORMS OF LEUKEMIA AND OTHER CANCERS THAT OVEREXPRESS RNA BINDING PROTEIN FXR1
#542TARGETING LIGAND AND USE THEREOF
#543DOSING OF MUSCLE TARGETING COMPLEXES FOR TREATING DYSTROPHINOPATHIES
#544LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY
#545LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#546IRAP INHIBITORS FOR USE IN THE TREATMENT OF INFLAMMATORY DISEASES
#547COMBINED TARGETING OF STAT3 AND ULKI TO TREAT GLIOBLASTOMA
#548Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#549ANTIVIRAL ANTISENSE OLIGONUCLEOTIDE
#550RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS
#551COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS
#552DELIVERY OF ANITSENSE OLIGOMERS BY MIRROR IMAGE PEPTIDES
#553HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#554Engineered Guide RNAs and Polynucleotides
#555ANTISENSE COMPOUNDS AND METHODS FOR TARGETING CUG REPEATS
#556COMPOSITIONS AND METHODS FOR TREATING TDP-43 PROTEINOPATHY
#557NEURODEGENERATIVE DISORDERS
#558COMPOUND AND LIPID COMPOSITION
#559Methods and Compositions for Treating Cancers and Enhancing Therapeutic Immunity by Selectively Reducing Immunomodulatory M2 Monocytes
#560METHOD OF TREATMENT FOR OPTIC ATROPHY
#561MOLECULAR THERAPEUTICS FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY AND HEART FAILURE ASSOCIATED WITH MYBPC3 GENE MUTATIONS
#562COMPOSITIONS AND METHODS FOR THE TREATMENT OF PCDH19 RELATED DISORDERS
#563TREATMENT OF COMPLEMENT-MEDIATED DISORDERS
#564BLOCK COPOLYMERS AND USES THEREOF
#565POLY-GA PROTEINS IN ALZHEIMER’S DISEASE
#566PARN AS A BIOMARKER AND THERAPEUTIC TARGET
#567PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV
#568Means and Methods for Chronic Wound Healing
#569PEPTIDE HAVING INDEPENDENTLY STABILIZED HYDROPHOBIC ALPHA HELIX, PEPTIDE COMPLEX COMPRISING SAME AND USES THEREOF
#570METHODS AND COMPOSITIONS FOR TARGETING SV2 PROTEINS FOR IMMUNE REGULATION
#571Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#572IMMUNOTHERAPIES FOR THE TREATMENT OF CANCER
#573METHODS AND COMPOSITIONS FOR TREATING EPILEPSY
#574TIS-L TARGETING ANTIVIRAL ANTISENSE OLIGONUCLEOTIDE WITH ABILITY TO INHIBIT VIRAL REPLICATION OF SARS-COV-2
#575THERAPEUTIC TREATMENT FOR FRAGILE X-ASSOCIATED DISORDER
#576FOLDING OLIGONUCLEOTIDES
#577OLIGONUCLEOTIDES FOR TARGETING COMPLEMENT C5
#578SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
#579COMPOSITIONS AND METHODS FOR SKIPPING EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY
#580POLYMER NANOPARTICLE AND DNA NANOSTRUCTURE COMPOSITIONS AND METHODS FOR NON-VIRAL DELIVERY
#581ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN
#582SYSTEMS AND METHODS FOR DETERMINING EFFECTS OF THERAPIES AND GENETIC VARIATION ON POLYADENYLATION SITE SELECTION
#583RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S SYNDROME
#584MODIFIED AAV CONSTRUCTS AND USES THEREOF
#585RNAi TARGETING HNRNPH2 MISSENSE MUTATIONS FOR TREATMENT OF BAIN SYNDROME
#586CORRECTION OF SPLICING MUTATIONS CAUSING PRIMARY CILIARY DYSKINESIA USING OLIGONUCLEOTIDES
#587COMPOSITIONS AND METHODS FOR MODULATING NLRP3 OR NLRP1 EXPRESSION
#588MUC5B-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR MODULATING MUCIN EXPRESSION
#589NOVEL RNA TRANSCRIPT
#590INTEGRIN TARGETING LIGANDS FOR OCULAR DELIVERY OF RNAI COMPOUNDS
#591PREVENTIVE OR THERAPEUTIC AGENT FOR BENIGN ADULT FAMILIAL MYOCLONIC EPILEPSY
#592MODELS OF TAUOPATHY
#593Muscle targeting complexes and uses thereof for treating dystrophinopathies
#594UNC13A ANTISENSE OLIGONUCLEOTIDES
#595ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#596IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#597COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#598AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#599THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#600SGF29 AS A TARGET FOR HOX/MYC DRIVEN CANCERS