109196 ⎘
Structure or type of the nucleic acid; Chemical structure; Nature of the modification; Conjugate Lipophilic moiety, e.g. cholesterol
PHARMACEUTICAL COMPOSITION FOR TREATING SPINOCEREBELLAR ATAXIA
#2CORONAVIRUS IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3Enhancing Oligonucleotide Immunomodulatory Activity through Dianophore Long-Lasting Modification: Methods and Applications
#4COMPOSITIONS AND METHODS FOR PROGRAMMED DEATH LIGAND RECEPTOR (PD-L1) EXPRESSION
#5COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#6PLIN1 RNAi INTERFERENCE AGENTS
#7COMPOSITIONS AND METHODS FOR DELIVERING A MACROMOLECULE TO A CELL
#8USE OF MIR-15A-5P IN TREATMENT OF FUNDUS OCULI DISEASE
#9MODIFIED RNA FOR INCREASING PROTEIN EXPRESSION
#10IMMUNOMODULATING POLYNUCLEOTIDES, ANTIBODY CONJUGATES THEREOF, AND METHODS OF THEIR USE
#11Methods for Preventing Cardiovascular Events Through Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Reduction
#12POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF
#13C-MYC-TARGETING CHARGE-ALTERING RELEASABLE TRANSPORTERS AS ANTI-TUMOR AGENTS FOR BREAST CANCER THERAPY
#14DNA-RNA HETERODUPLEX TARGETING ANDROGEN RECEPTOR
#15NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#16Methods for Directing Lipid Nanoparticles in Vivo
#17Use of a Janus Kinase Inhibitor and a Telomerase Inhibitor for the Treatment of Myeloproliferative Neoplasms
#18NUCLEIC ACID CARRIER AND METHOD FOR ADMINISTERING NUCLEIC ACID
#19OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF
#20LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO ADIPOSE TISSUE
#21EXTRACELLULAR VESICLE COMPRISING A BIOLOGICALLY ACTIVE MOLECULE AND A DUAL CLEAVABLE LINKER
#22REGULATION OF ACTIVITY OF RNAI MOLECULES
#23Synthetic Nanostructures Including Nucleic Acids and/or Other Entities
#24COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#25COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#26BRANCHED LIPID CONJUGATES OF siRNA FOR SPECIFIC TISSUE DELIVERY
#27COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#28SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#29RNA INTERFERENCE OLIGONUCLEOTIDES FOR INHIBITING PERINEURONAL NETWORK FORMATION
#30COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
#31COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#32Ligand-Modified Oligonucleotides
#33CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#34MODIFIED NUCLEIC ACID CONJUGATES
#35SIRNA MOLECULE AGAINST HUMAN TENASCIN-C (TNC) AND A PHARMACEUTICAL COMPOSITION COMPRISING IT
#36Conjugated Antisense Compounds and Their Use
#3717ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#38BBB-CROSSING LIPID LIGAND OF HETERO NUCLEIC ACID
#39TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#40Conjugated Antisense Compounds for Use in Therapy
#41APTAMER-BASED POLLUTANT PROTECTION
#42MUCIN-5B (MUC5B) TARGETED SIRNA AND ANTISENSE OLIGONUCLEOTIDES AND METHODS OF USE THEREOF
#43CONJUGATES FOR TISSUE-SPECIFIC OLIGONUCLEOTIDE DELIVERY
#44SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY
#45HIGH-AFFINITY THROMBIN APTAMERS AND METHODS OF USE
#46TREATMENT OF CARDIOVASCULAR DISEASE
#47OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#48CERTAIN DUX4 INHIBITORS AND METHODS OF USE THEREOF
#49COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#50STAT3 TARGETING OLIGONUCLEOTIDES AND USES THEREOF
#51Biradial Spherical Nucleic Acids
#52ACTIN-BINDING LIM PROTEIN 3 (ABLIM3) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#53MODIFIED DOUBLE STRANDED OLIGONUCLEOTIDES
#54OLIGONUCLEOTIDES FOR PRNP MODULATION
#55POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF
#56SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#57ANTI-CANCER AGENTS
#58MSI2 AS A THERAPEUTIC TARGET FOR THE TREATMENT OF MYOTONIC DYSTROPHY
#59Ribonucleic Acids With 4'-Thio-Modified Nucleotides and Related Methods
#60XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#61DOUBLE-STRANDED RNA MOLECULE FOR ADMINISTRATION TO THE EYE
#62MODIFIED OLIGONUCLEOTIDES
#63OLIGONUCLEOTIDES CONJUGATES COMPRISING 7'-5'-ALPHA-ANOMERIC-BICYCLIC SUGAR NUCLEOSIDES
#64OVERSUBSCRIPTION SCHEDULING
#65Targeting Ligands For Therapeutic Compounds
#66LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO CNS TISSUE
#67IMMUNOSTIMULATORY COMPOSITIONS
#68BRANCHED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS
#69AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#70COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF ALPHA-1 ANTITRYPSIN
#71RNAi Agents of Modulating PLP1
#72COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#73KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#74NONCOVALENTLY BRANCHED OLIGONUCLEOTIDE COMPOSITIONS
#75FULLY STABILIZED ASYMMETRIC SIRNA
#76LIPOPHILIC OLIGONUCLEOTIDE CONJUGATES
#77TARGETED COMPOSITIONS
#78COMPOUNDS AND METHODS FOR MODULATING SMN2
#79ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREATMENT OF CARDIO-METABOLIC DISEASES
#80APTAMERS, PHARMACEUTICAL COMPOSITIONS THEREOF, AND METHODS FOR PREVENTING OR TREATING BCMA-ASSOCIATED DISEASES OR CONDITIONS
#81COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#82Microtubule Associated Protein Tau (MAPT) iRNA Agent Compositions and Methods of Use Thereof
#83NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#84NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#85ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF
#86COMPOSITIONS CONTAINING POLYNUCLEOTIDE AMPHIPHILES AND METHODS OF USE THEREOF
#87RNAi OLIGONUCLEOTIDE CONJUGATES
#88TETRAMOLECULAR PARALLEL G-QUADRUPLEX-FORMING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#89DNA ORIGAMI STRUCTURE AND PROTEIN NANOPORE CONSTRUCT
#90CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING
#91COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#92HEPARIN SULFATE BIOSYNTHESIS PATHWAY ENZYME IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#93COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND MOTOR BEHAVIOR
#94TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES
#95DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF
#96COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#97SGLT-2 TARGETING OLIGONUCLEOTIDES
#98TUNABLE REVERSIR TM COMPOUNDS
#99BIOACTIVE CONJUGATES FOR OLIGONUCLEOTIDE DELIVERY
#100APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1013-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#102OLIGONUCLEOTIDES FOR SNCA MODULATION
#103NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
#104STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#105LIPID-PEGYLATED COMPOUNDS, PREPARATIONS AND USES THEREOF
#106COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#107POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF
#108LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY
#109AGENTS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS
#110HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#111OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME
#112NUCLEIC ACID-BASED ASSEMBLY AND USES THEREOF
#113OLIGONUCLEOTIDES FOR SARS-CoV-2 MODULATION
#114NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#115OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION
#116iRNA Compositions and Methods for Targeting ANGPTL7
#117CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TREATING NEUROLOGICAL DISEASES
#118COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#119COMPOSITIONS AND METHODS FOR MODULATING PNPLA3 EXPRESSION
#120TUMOR DELIVERY OF DENDRITIC OLIGONUCLEOTIDES
#121COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#122MICRORNA-29 COMPOUNDS, COMPOSITIONS AND USES IN THERAPY
#123OLIGOMERIC COMPOUND FOR DYSTROPHIN RESCUE IN DMD PATIENTS THROUGHOUT SKIPPING OF EXON-51
#124LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#125EXTRAHEPATIC DELIVERY
#126ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CANCER
#127Compositions and methods for modulating apolipoprotein (a) expression
#128BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#129DNAZYMES TARGETING CELL WALL SYNTHESIS ENZYMES AND USES THEREOF
#130LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE
#131Double-Stranded Nucleic Acid Molecule for Treating Proliferative Vitreoretinopathy and Use Thereof
#132DISE-INDUCING SRNA-POLYPLEXES AND SRNA-LIPOPOLYPLEXES AND METHODS OF USING THE SAME TO TREAT CANCER
#133VON WILLEBRAND FACTOR (VWF)-TARGETING AGENTS AND METHODS OF USING THE SAME
#134Compositions and Methods for Silencing MYOC Expression
#135OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#136CHEMICALLY MODIFIED OLIGONUCLEOTIDES
#137LEUCINE-RICH REPEAT KINASE 2 (LRRK2) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#138iRNA Compositions and Methods for Silencing Filamin A (FLNA)
#139NEW CONJUGATED NUCLEIC ACID MOLECULES AND THEIR USES
#140INSULIN-LIKE GROWTH FACTOR BINDING PROTEIN, ACID LABILE SUBUNIT (IGFALS) AND INSULIN-LIKE GROWTH FACTOR 1 (IGF-1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#141ATXN2 IRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING ATXN2-ASSOCIATED NEURODEGENERATIVE DISEASES
#142BRANCHED OLIGONUCLEOTIDES
#143TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS
#144OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION
#145LIPID CONJUGATION FOR TARGETING NEURONS OF THE CENTRAL NERVOUS SYSTEM
#146IL-15 Conjugates and Uses Thereof
#147Conjugated antisense compounds and their use
#148SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#149MIRNA INHIBITORS FOR PREVENTING AND TREATING ANEURYSMS, HYPERTENSION, ARDS AND OTHER DISEASES ASSOCIATED WITH ENDOTHELIAL DYSFUNCTION
#150LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF INFLAMMATORY DISEASES
#151SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
#152COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#153SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION FACTOR 6 (STAT6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#154EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
#155FATTY ACID CONJUGATES OF NUCLEIC ACIDS
#156CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#157HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#158Compositions for Inhibiting Growth of Targeted Cells
#159MODULATING APOLIPOPROTEIN (A) EXPRESSION
#160iRNA COMPOSITIONS AND METHODS FOR SILENCING CHITINASE 3-LIKE PROTEIN 1/YKL-40 (CHI3L1/YKL-40) PROTEIN
#161ELONGATION OF VERY LONG CHAIN FATTY ACIDS PROTEIN 1 (ELOVL1) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#162NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE
#163STEAROYL-COA DESATURASE 5 (SCD5) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#164ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#165TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#166MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#167OLIGONUCLEOTIDES TARGETING S6K1
#168KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#169Non-liposomal systems for nucleic acid delivery
#170DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS
#171OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#172ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#173DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES
#174Skeletal Muscle Delivery Platforms and Methods of Use
#175COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#176MODIFIED GUIDE RNAS FOR CRISPR GENOME EDITING
#177Conjugated Antisense Compounds for Use in Therapy
#178CHIMERIC DOUBLE-STRANDED NUCLEIC ACID
#179OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME
#180PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#181GLYCOGEN SYNTHASE KINASE 3 ALPHA (GSK3 ALPHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#182PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#183Lipid-pegylated compounds, preparations and uses thereof
#184COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
#185iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)
#186MODIFIED HETERO NUCLEIC ACIDS
#187COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#188SUBSTANCES AND METHODS FOR TREATING DYSTROPHIC EPIDERMOLYSIS BULLOSA
#189COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES
#190POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF
#191COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#192COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#193RNAi AGENT TARGETING MYD88 AND USE THEREOF
#194ANTISENSE OLIGOMERS TARGETING PCSK9
#195CONJUGATED OLIGONUCLEOTIDES
#196DIPEPTIDYL PEPTIDASE 4 (DPP4) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#197Lipids and compositions for the delivery of therapeutics
#198Oligomers and oligomer conjugates
#199RNAi agents for inhibiting expression of Superoxide Dismutase 1 (SOD1), compositions thereof, and methods of use
#200GALNAC COMPOSITIONS FOR IMPROVING SIRNA BIOAVAILABILITY
#201Extrahepatic delivery
#202TREATMENT OF FUCHS' ENDOTHELIAL CORNEAL DYSTROPHY
#203COMPOSITIONS AND METHODS FOR INHIBITING SNCA EXPRESSION
#204COMPOSITIONS AND METHODS FOR INHIBITING MAPT EXPRESSION
#205EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#206G PROTEIN-COUPLED RECEPTOR 75 (GPR75) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#207COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#208NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#209COMPOUNDS AND METHODS FOR MODULATING PMP22
#210Effect of Fuel Doping in ICF Targets
#211OLIGONUCLEIC ACID CONJUGATE
#212ENDOSOMAL ESCAPE DOMAINS FOR DELIVERY OF MACROMOLECULES INTO CELLS
#213METHODS AND COMPOSITIONS FOR MACROPHAGE POLARIZATION
#214SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#215COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES
#216RNAI AGENTS FOR HEPATITIS B VIRUS INFECTION
#217TREATMENT OF SKIN DISEASES AND DISORDERS USING INHIBITORS OF KALLIKREIN-RELATED PEPTIDASES (KLK)
#218SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#219Amphiregulin gene-specific double-stranded oligonucleotide and composition for preventing and treating fibrosis-related diseases and respiratory diseases, comprising same
#220IRNA COMPOSITIONS AND METHODS FOR SILENCING GROWTH FACTOR RECEPTOR BOUND PROTEIN 10 (GRB10) OR GROWTH FACTOR RECEPTOR BOUND PROTEIN 14 (GRB14) IN THE LIVER
#221ANTISENSE RNA FOR TREATMENT OF SARS-ASSOCIATED CORONAVIRUS
#222Modified oligonucleotides
#223TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#224LOADING OF EXTRACELLULAR VESICLES THROUGH IMPARTING OF MECHANICAL SHEAR
#225COMPOSITIONS AND METHODS FOR SILENCING MYOC EXPRESSION
#226METHODS AND COMPOSITIONS OF BIOLOGICALLY ACTIVE AGENTS
#227Inhibition of lncExACT1 to Treat Heart Disease
#228RNAi COMPOSITIONS AND METHODS OF USE THEREOF FOR DELIVERY BY INHALATION
#229MUCOPENETRATING FORMULATIONS
#230siRNAs WITH VINYLPHOSPHONATE AT THE 5' END OF THE ANTISENSE STRAND
#231COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING COMPLEMENT COMPONENT C3-ASSOCIATED DISEASES
#232METHODS OF TREATING AND PREVENTING BACTERIAL INFECTIONS
#233Compositions and methods for inhibiting expression of transthyretin
#234APTAMER FOR IL-21 AND USE THEREOF
#235LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS
#236COMPOSITIONS AND METHODS FOR TREATING HYPERTRIGLYCERIDEMIA
#237MONOCYTE-SPECIFIC APTAMERS AND USES THEREOF FOR ENHANCING DRUG DELIVERY TO CANCER
#238SINGLE-STRANDED OLIGONUCLEOTIDE
#239AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#240Compositions and methods of treating muscle atrophy and myotonic dystrophy
#241Compositions and methods of treating muscle atrophy and myotonic dystrophy
#242CYTOTOXIC T-LYMPHOCYTE BINDING APTAMERS
#243BISPECIFIC PERSONALIZED APTAMERS
#244TRANSMEMBRANE SERINE PROTEASE 2 (TMPRSS2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#245NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#246APOLIPOPROTEIN E (APOE) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#247Ribonucleic acids with 4′-thio-modified nucleotides and related methods
#248Immunostimulatory compositions
#249HETERONUCLEIC ACID CONTAINING MORPHOLINO NUCLEIC ACID
#250Aptamer-Engineered Natural Killer Cells for Cell-Specific Adaptive Immunotherapy
#251COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION
#252ANTISENSE OLIGONUCLEOTIDE OF CALM2
#253COMPOUND COMPRISING A NUCLEIC ACID AND A HALF-LIFE EXTENSION MOTIF
#254COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#255OXIDIZED TUMOR CELL LYSATES ENCAPSULATED IN LIPOSOMAL SPHERICAL NUCLEIC ACIDS AS POTENT CANCER IMMUNOTHERAPEUTICS
#256SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY
#257RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#258ALPHA-2A ADRENERGIC RECEPTOR (ADRA2A) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#259COMPOSITIONS AND METHODS FOR SILENCING VEGF-A EXPRESSION
#260ANGIOTENSIN-CONVERTING ENZYME 2 (ACE2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#261OLIGONUCLEOTIDES CONJUGATES COMPRISING 7'-5'-ALPHA-ANOMERIC-BICYCLIC SUGAR NUCLEOSIDES
#262LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#263RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#264USP10 TARGETED SELF-DELIVERABLE SIRNA COMPOSITIONS AND METHODS FOR PREVENTING OR INHIBITING FIBROSIS AND/OR SCARRING
#265COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#266HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#267Targeted compositions
#268Nucleic acid and other compositions and methods for the modulation of cell membranes
#269CONDITIONAL-siRNAS AND USES THEREOF IN TREATING CARDIAC HYPERTROPHY
#270MICRORNA COMPOSITIONS AND METHODS OF USE
#271ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS
#272STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#273PRODUCTS AND COMPOSITIONS
#274MIR-149-3P AND METHOD FOR TREATING METABOLIC DISEASE USING THE SAME
#275APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2764′-phosphate analogs and oligonucleotides comprising the same
#277ATAXIN3 (ATXN3) RNAI AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#278METHOD AND COMPOSITION FOR MEASUREMENT OF NITRIC OXIDE
#279COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#280Compositions and Methods Comprising a TTR Guide RNA and a Polynucleotide Encoding an RNA-Guided DNA Binding Agent
#281SMALL RIBOSOMAL PROTEIN SUBUNIT 25 (RPS25) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#282Tunable Reversir™ compounds
#283MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#284Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#285Oligonucleotides for SARS-CoV-2 modulation
#286RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#287PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#288Compositions and methods for inhibiting gene expression of alpha-1 antitrypsin
#289CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY
#290COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#291MODIFIED iRNA AGENTS
#292OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF
#293NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#294ASYMMETRIC SIRNA INHIBITING EXPRESSION OF PD-1
#295Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof
#296HUNTINGTIN (HTT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#297PPM1A INHIBITORS AND METHODS OF USING SAME
#298Dynamic pharmacokinetic-modifying anchors
#299Compositions and methods for modulating PNPLA3 expression
#300ANTISENSE OLIGONUCLEOTIDE CAPABLE OF ALTERING SPLICING OF DUX4 pre-mRNA