ClassID:

109196

C12N2310/3515 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Chemical structure; Nature of the modification; Conjugate Lipophilic moiety, e.g. cholesterol

Recent Application in this class:
#1
20260159839
2026-06-11

PHARMACEUTICAL COMPOSITION FOR TREATING SPINOCEREBELLAR ATAXIA

#2
20260159837
2026-06-11

CORONAVIRUS IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#3
20260146254
2026-05-28

Enhancing Oligonucleotide Immunomodulatory Activity through Dianophore Long-Lasting Modification: Methods and Applications

#4
20260146253
2026-05-28

COMPOSITIONS AND METHODS FOR PROGRAMMED DEATH LIGAND RECEPTOR (PD-L1) EXPRESSION

#5
20260146252
2026-05-28

COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS

#6
20260139257
2026-05-21

PLIN1 RNAi INTERFERENCE AGENTS

#7
20260137807
2026-05-21

COMPOSITIONS AND METHODS FOR DELIVERING A MACROMOLECULE TO A CELL

#8
20260125674
2026-05-07

USE OF MIR-15A-5P IN TREATMENT OF FUNDUS OCULI DISEASE

#9
20260109977
2026-04-23

MODIFIED RNA FOR INCREASING PROTEIN EXPRESSION

#10
20260109728
2026-04-23

IMMUNOMODULATING POLYNUCLEOTIDES, ANTIBODY CONJUGATES THEREOF, AND METHODS OF THEIR USE

#11
20260108631
2026-04-23

Methods for Preventing Cardiovascular Events Through Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Reduction

#12
20260103715
2026-04-16

POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF

#13
20260103709
2026-04-16

C-MYC-TARGETING CHARGE-ALTERING RELEASABLE TRANSPORTERS AS ANTI-TUMOR AGENTS FOR BREAST CANCER THERAPY

#14
20260092282
2026-04-02

DNA-RNA HETERODUPLEX TARGETING ANDROGEN RECEPTOR

#15
20260092280
2026-04-02

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#16
20260078381
2026-03-19

Methods for Directing Lipid Nanoparticles in Vivo

#17
20260078379
2026-03-19

Use of a Janus Kinase Inhibitor and a Telomerase Inhibitor for the Treatment of Myeloproliferative Neoplasms

#18
20260077057
2026-03-19

NUCLEIC ACID CARRIER AND METHOD FOR ADMINISTERING NUCLEIC ACID

#19
20260076989
2026-03-19

OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF

#20
20260071223
2026-03-12

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO ADIPOSE TISSUE

#21
20260055411
2026-02-26

EXTRACELLULAR VESICLE COMPRISING A BIOLOGICALLY ACTIVE MOLECULE AND A DUAL CLEAVABLE LINKER

#22
20260049309
2026-02-19

REGULATION OF ACTIVITY OF RNAI MOLECULES

#23
20260048010
2026-02-19

Synthetic Nanostructures Including Nucleic Acids and/or Other Entities

#24
20260035695
2026-02-05

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION

#25
20260027146
2026-01-29

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#26
20260015614
2026-01-15

BRANCHED LIPID CONJUGATES OF siRNA FOR SPECIFIC TISSUE DELIVERY

#27
20260007766
2026-01-08

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#28
20260002155
2026-01-01

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#29
20250388899
2025-12-25

RNA INTERFERENCE OLIGONUCLEOTIDES FOR INHIBITING PERINEURONAL NETWORK FORMATION

#30
20250376682
2025-12-11

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN

#31
20250375388
2025-12-11

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#32
20250353872
2025-11-20

Ligand-Modified Oligonucleotides

#33
20250346899
2025-11-13

CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE

#34
20250346891
2025-11-13

MODIFIED NUCLEIC ACID CONJUGATES

#35
20250340875
2025-11-06

SIRNA MOLECULE AGAINST HUMAN TENASCIN-C (TNC) AND A PHARMACEUTICAL COMPOSITION COMPRISING IT

#36
20250333741
2025-10-30

Conjugated Antisense Compounds and Their Use

#37
20250333737
2025-10-30

17ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#38
20250333736
2025-10-30

BBB-CROSSING LIPID LIGAND OF HETERO NUCLEIC ACID

#39
20250333732
2025-10-30

TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS

#40
20250319116
2025-10-16

Conjugated Antisense Compounds for Use in Therapy

#41
20250313847
2025-10-09

APTAMER-BASED POLLUTANT PROTECTION

#42
20250313840
2025-10-09

MUCIN-5B (MUC5B) TARGETED SIRNA AND ANTISENSE OLIGONUCLEOTIDES AND METHODS OF USE THEREOF

#43
20250313839
2025-10-09

CONJUGATES FOR TISSUE-SPECIFIC OLIGONUCLEOTIDE DELIVERY

#44
20250312490
2025-10-09

SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY

#45
20250304973
2025-10-02

HIGH-AFFINITY THROMBIN APTAMERS AND METHODS OF USE

#46
20250304966
2025-10-02

TREATMENT OF CARDIOVASCULAR DISEASE

#47
20250297942
2025-09-25

OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN

#48
20250297251
2025-09-25

CERTAIN DUX4 INHIBITORS AND METHODS OF USE THEREOF

#49
20250295805
2025-09-25

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#50
20250290071
2025-09-18

STAT3 TARGETING OLIGONUCLEOTIDES AND USES THEREOF

#51
20250283095
2025-09-11

Biradial Spherical Nucleic Acids

#52
20250283079
2025-09-11

ACTIN-BINDING LIM PROTEIN 3 (ABLIM3) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#53
20250283071
2025-09-11

MODIFIED DOUBLE STRANDED OLIGONUCLEOTIDES

#54
20250277221
2025-09-04

OLIGONUCLEOTIDES FOR PRNP MODULATION

#55
20250276091
2025-09-04

POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF

#56
20250276001
2025-09-04

SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#57
20250270560
2025-08-28

ANTI-CANCER AGENTS

#58
20250270549
2025-08-28

MSI2 AS A THERAPEUTIC TARGET FOR THE TREATMENT OF MYOTONIC DYSTROPHY

#59
20250257090
2025-08-14

Ribonucleic Acids With 4'-Thio-Modified Nucleotides and Related Methods

#60
20250250572
2025-08-07

XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#61
20250250571
2025-08-07

DOUBLE-STRANDED RNA MOLECULE FOR ADMINISTRATION TO THE EYE

#62
20250250568
2025-08-07

MODIFIED OLIGONUCLEOTIDES

#63
20250250565
2025-08-07

OLIGONUCLEOTIDES CONJUGATES COMPRISING 7'-5'-ALPHA-ANOMERIC-BICYCLIC SUGAR NUCLEOSIDES

#64
20250243489
2025-07-31

OVERSUBSCRIPTION SCHEDULING

#65
20250243485
2025-07-31

Targeting Ligands For Therapeutic Compounds

#66
20250223597
2025-07-10

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO CNS TISSUE

#67
20250215439
2025-07-03

IMMUNOSTIMULATORY COMPOSITIONS

#68
20250215432
2025-07-03

BRANCHED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS

#69
20250207137
2025-06-26

AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME

#70
20250197861
2025-06-19

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF ALPHA-1 ANTITRYPSIN

#71
20250197858
2025-06-19

RNAi Agents of Modulating PLP1

#72
20250195676
2025-06-19

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#73
20250188475
2025-06-12

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#74
20250188471
2025-06-12

NONCOVALENTLY BRANCHED OLIGONUCLEOTIDE COMPOSITIONS

#75
20250188458
2025-06-12

FULLY STABILIZED ASYMMETRIC SIRNA

#76
20250188455
2025-06-12

LIPOPHILIC OLIGONUCLEOTIDE CONJUGATES

#77
20250179496
2025-06-05

TARGETED COMPOSITIONS

#78
20250179493
2025-06-05

COMPOUNDS AND METHODS FOR MODULATING SMN2

#79
20250179485
2025-06-05

ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREATMENT OF CARDIO-METABOLIC DISEASES

#80
20250171787
2025-05-29

APTAMERS, PHARMACEUTICAL COMPOSITIONS THEREOF, AND METHODS FOR PREVENTING OR TREATING BCMA-ASSOCIATED DISEASES OR CONDITIONS

#81
20250171785
2025-05-29

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE

#82
20250171777
2025-05-29

Microtubule Associated Protein Tau (MAPT) iRNA Agent Compositions and Methods of Use Thereof

#83
20250171544
2025-05-29

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#84
20250152726
2025-05-15

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#85
20250136992
2025-05-01

ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF

#86
20250134992
2025-05-01

COMPOSITIONS CONTAINING POLYNUCLEOTIDE AMPHIPHILES AND METHODS OF USE THEREOF

#87
20250122500
2025-04-17

RNAi OLIGONUCLEOTIDE CONJUGATES

#88
20250122496
2025-04-17

TETRAMOLECULAR PARALLEL G-QUADRUPLEX-FORMING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES

#89
20250101415
2025-03-27

DNA ORIGAMI STRUCTURE AND PROTEIN NANOPORE CONSTRUCT

#90
20250099497
2025-03-27

CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING

#91
20250084418
2025-03-13

COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION

#92
20250084417
2025-03-13

HEPARIN SULFATE BIOSYNTHESIS PATHWAY ENZYME IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#93
20250075215
2025-03-06

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND MOTOR BEHAVIOR

#94
20250075211
2025-03-06

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES

#95
20250064940
2025-02-27

DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF

#96
20250064936
2025-02-27

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#97
20250059539
2025-02-20

SGLT-2 TARGETING OLIGONUCLEOTIDES

#98
20250059536
2025-02-20

TUNABLE REVERSIR TM COMPOUNDS

#99
20250059533
2025-02-20

BIOACTIVE CONJUGATES FOR OLIGONUCLEOTIDE DELIVERY

#100
20250051765
2025-02-13

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#101
20250043289
2025-02-06

3-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#102
20250043284
2025-02-06

OLIGONUCLEOTIDES FOR SNCA MODULATION

#103
20250034571
2025-01-30

NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY

#104
20250034570
2025-01-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#105
20250027091
2025-01-23

LIPID-PEGYLATED COMPOUNDS, PREPARATIONS AND USES THEREOF

#106
20250019699
2025-01-16

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE

#107
20250019409
2025-01-16

POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF USE THEREOF

#108
20250018045
2025-01-16

LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY

#109
20250011815
2025-01-09

AGENTS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS

#110
20250011776
2025-01-09

HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#111
20250011359
2025-01-09

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME

#112
20240425867
2024-12-26

NUCLEIC ACID-BASED ASSEMBLY AND USES THEREOF

#113
20240425860
2024-12-26

OLIGONUCLEOTIDES FOR SARS-CoV-2 MODULATION

#114
20240424105
2024-12-26

NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS

#115
20240417723
2024-12-19

OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION

#116
20240409943
2024-12-12

iRNA Compositions and Methods for Targeting ANGPTL7

#117
20240409933
2024-12-12

CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TREATING NEUROLOGICAL DISEASES

#118
20240401060
2024-12-05

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#119
20240401059
2024-12-05

COMPOSITIONS AND METHODS FOR MODULATING PNPLA3 EXPRESSION

#120
20240401042
2024-12-05

TUMOR DELIVERY OF DENDRITIC OLIGONUCLEOTIDES

#121
20240401038
2024-12-05

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION

#122
20240390410
2024-11-28

MICRORNA-29 COMPOUNDS, COMPOSITIONS AND USES IN THERAPY

#123
20240368591
2024-11-07

OLIGOMERIC COMPOUND FOR DYSTROPHIN RESCUE IN DMD PATIENTS THROUGHOUT SKIPPING OF EXON-51

#124
20240360448
2024-10-31

LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF

#125
20240358738
2024-10-31

EXTRAHEPATIC DELIVERY

#126
20240352462
2024-10-24

ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CANCER

#127
20240352455
2024-10-24

Compositions and methods for modulating apolipoprotein (a) expression

#128
20240344066
2024-10-17

BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#129
20240336923
2024-10-10

DNAZYMES TARGETING CELL WALL SYNTHESIS ENZYMES AND USES THEREOF

#130
20240327834
2024-10-03

LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE

#131
20240327833
2024-10-03

Double-Stranded Nucleic Acid Molecule for Treating Proliferative Vitreoretinopathy and Use Thereof

#132
20240327830
2024-10-03

DISE-INDUCING SRNA-POLYPLEXES AND SRNA-LIPOPOLYPLEXES AND METHODS OF USING THE SAME TO TREAT CANCER

#133
20240318178
2024-09-26

VON WILLEBRAND FACTOR (VWF)-TARGETING AGENTS AND METHODS OF USING THE SAME

#134
20240318175
2024-09-26

Compositions and Methods for Silencing MYOC Expression

#135
20240309369
2024-09-19

OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN

#136
20240301430
2024-09-12

CHEMICALLY MODIFIED OLIGONUCLEOTIDES

#137
20240301426
2024-09-12

LEUCINE-RICH REPEAT KINASE 2 (LRRK2) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#138
20240301418
2024-09-12

iRNA Compositions and Methods for Silencing Filamin A (FLNA)

#139
20240294926
2024-09-05

NEW CONJUGATED NUCLEIC ACID MOLECULES AND THEIR USES

#140
20240294911
2024-09-05

INSULIN-LIKE GROWTH FACTOR BINDING PROTEIN, ACID LABILE SUBUNIT (IGFALS) AND INSULIN-LIKE GROWTH FACTOR 1 (IGF-1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#141
20240294906
2024-09-05

ATXN2 IRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING ATXN2-ASSOCIATED NEURODEGENERATIVE DISEASES

#142
20240293550
2024-09-05

BRANCHED OLIGONUCLEOTIDES

#143
20240287519
2024-08-29

TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS

#144
20240287514
2024-08-29

OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION

#145
20240287512
2024-08-29

LIPID CONJUGATION FOR TARGETING NEURONS OF THE CENTRAL NERVOUS SYSTEM

#146
20240287151
2024-08-29

IL-15 Conjugates and Uses Thereof

#147
20240279664
2024-08-22

Conjugated antisense compounds and their use

#148
20240271144
2024-08-15

SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#149
20240271132
2024-08-15

MIRNA INHIBITORS FOR PREVENTING AND TREATING ANEURYSMS, HYPERTENSION, ARDS AND OTHER DISEASES ASSOCIATED WITH ENDOTHELIAL DYSFUNCTION

#150
20240271130
2024-08-15

LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF INFLAMMATORY DISEASES

#151
20240255880
2024-08-01

SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT

#152
20240254493
2024-08-01

COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION

#153
20240254484
2024-08-01

SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION FACTOR 6 (STAT6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#154
20240254481
2024-08-01

EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6

#155
20240247274
2024-07-25

FATTY ACID CONJUGATES OF NUCLEIC ACIDS

#156
20240247260
2024-07-25

CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE

#157
20240240182
2024-07-18

HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#158
20240229033
2024-07-11

Compositions for Inhibiting Growth of Targeted Cells

#159
20240218361
2024-07-04

MODULATING APOLIPOPROTEIN (A) EXPRESSION

#160
20240209374
2024-06-27

iRNA COMPOSITIONS AND METHODS FOR SILENCING CHITINASE 3-LIKE PROTEIN 1/YKL-40 (CHI3L1/YKL-40) PROTEIN

#161
20240209373
2024-06-27

ELONGATION OF VERY LONG CHAIN FATTY ACIDS PROTEIN 1 (ELOVL1) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#162
20240200081
2024-06-20

NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE

#163
20240200077
2024-06-20

STEAROYL-COA DESATURASE 5 (SCD5) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#164
20240200075
2024-06-20

ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#165
20240200061
2024-06-20

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES

#166
20240189339
2024-06-13

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#167
20240182904
2024-06-06

OLIGONUCLEOTIDES TARGETING S6K1

#168
20240182902
2024-06-06

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#169
20240182895
2024-06-06

Non-liposomal systems for nucleic acid delivery

#170
20240182892
2024-06-06

DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS

#171
20240175801
2024-05-30

OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN

#172
20240175030
2024-05-30

ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#173
20240175024
2024-05-30

DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES

#174
20240175019
2024-05-30

Skeletal Muscle Delivery Platforms and Methods of Use

#175
20240175017
2024-05-30

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#176
20240167029
2024-05-23

MODIFIED GUIDE RNAS FOR CRISPR GENOME EDITING

#177
20240165146
2024-05-23

Conjugated Antisense Compounds for Use in Therapy

#178
20240158790
2024-05-16

CHIMERIC DOUBLE-STRANDED NUCLEIC ACID

#179
20240150391
2024-05-09

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME

#180
20240148773
2024-05-09

PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#181
20240132895
2024-04-25

GLYCOGEN SYNTHASE KINASE 3 ALPHA (GSK3 ALPHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#182
20240124882
2024-04-18

PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#183
20240117362
2024-04-11

Lipid-pegylated compounds, preparations and uses thereof

#184
20240117351
2024-04-11

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM

#185
20240117349
2024-04-11

iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)

#186
20240117346
2024-04-11

MODIFIED HETERO NUCLEIC ACIDS

#187
20240115679
2024-04-11

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#188
20240110181
2024-04-04

SUBSTANCES AND METHODS FOR TREATING DYSTROPHIC EPIDERMOLYSIS BULLOSA

#189
20240110180
2024-04-04

COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES

#190
20240102020
2024-03-28

POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF

#191
20240093201
2024-03-21

COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS

#192
20240093199
2024-03-21

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE

#193
20240093188
2024-03-21

RNAi AGENT TARGETING MYD88 AND USE THEREOF

#194
20240084307
2024-03-14

ANTISENSE OLIGOMERS TARGETING PCSK9

#195
20240084297
2024-03-14

CONJUGATED OLIGONUCLEOTIDES

#196
20240067972
2024-02-29

DIPEPTIDYL PEPTIDASE 4 (DPP4) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#197
20240042039
2024-02-08

Lipids and compositions for the delivery of therapeutics

#198
20240035032
2024-02-01

Oligomers and oligomer conjugates

#199
20240026363
2024-01-25

RNAi agents for inhibiting expression of Superoxide Dismutase 1 (SOD1), compositions thereof, and methods of use

#200
20240018523
2024-01-18

GALNAC COMPOSITIONS FOR IMPROVING SIRNA BIOAVAILABILITY

#201
20240009225
2024-01-11

Extrahepatic delivery

#202
20240002849
2024-01-04

TREATMENT OF FUCHS' ENDOTHELIAL CORNEAL DYSTROPHY

#203
20230416743
2023-12-28

COMPOSITIONS AND METHODS FOR INHIBITING SNCA EXPRESSION

#204
20230416742
2023-12-28

COMPOSITIONS AND METHODS FOR INHIBITING MAPT EXPRESSION

#205
20230399659
2023-12-14

EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES

#206
20230392156
2023-12-07

G PROTEIN-COUPLED RECEPTOR 75 (GPR75) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#207
20230390321
2023-12-07

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#208
20230381319
2023-11-30

NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS

#209
20230374519
2023-11-23

COMPOUNDS AND METHODS FOR MODULATING PMP22

#210
20230374511
2023-11-23

Effect of Fuel Doping in ICF Targets

#211
20230372505
2023-11-23

OLIGONUCLEIC ACID CONJUGATE

#212
20230372491
2023-11-23

ENDOSOMAL ESCAPE DOMAINS FOR DELIVERY OF MACROMOLECULES INTO CELLS

#213
20230365971
2023-11-16

METHODS AND COMPOSITIONS FOR MACROPHAGE POLARIZATION

#214
20230365965
2023-11-16

SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#215
20230357774
2023-11-09

COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES

#216
20230355651
2023-11-09

RNAI AGENTS FOR HEPATITIS B VIRUS INFECTION

#217
20230340488
2023-10-26

TREATMENT OF SKIN DISEASES AND DISORDERS USING INHIBITORS OF KALLIKREIN-RELATED PEPTIDASES (KLK)

#218
20230340473
2023-10-26

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#219
20230332154
2023-10-19

Amphiregulin gene-specific double-stranded oligonucleotide and composition for preventing and treating fibrosis-related diseases and respiratory diseases, comprising same

#220
20230332147
2023-10-19

IRNA COMPOSITIONS AND METHODS FOR SILENCING GROWTH FACTOR RECEPTOR BOUND PROTEIN 10 (GRB10) OR GROWTH FACTOR RECEPTOR BOUND PROTEIN 14 (GRB14) IN THE LIVER

#221
20230323353
2023-10-12

ANTISENSE RNA FOR TREATMENT OF SARS-ASSOCIATED CORONAVIRUS

#222
20230304008
2023-09-28

Modified oligonucleotides

#223
20230304002
2023-09-28

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES

#224
20230301917
2023-09-28

LOADING OF EXTRACELLULAR VESICLES THROUGH IMPARTING OF MECHANICAL SHEAR

#225
20230295622
2023-09-21

COMPOSITIONS AND METHODS FOR SILENCING MYOC EXPRESSION

#226
20230295617
2023-09-21

METHODS AND COMPOSITIONS OF BIOLOGICALLY ACTIVE AGENTS

#227
20230287427
2023-09-14

Inhibition of lncExACT1 to Treat Heart Disease

#228
20230287424
2023-09-14

RNAi COMPOSITIONS AND METHODS OF USE THEREOF FOR DELIVERY BY INHALATION

#229
20230287417
2023-09-14

MUCOPENETRATING FORMULATIONS

#230
20230272385
2023-08-31

siRNAs WITH VINYLPHOSPHONATE AT THE 5' END OF THE ANTISENSE STRAND

#231
20230272382
2023-08-31

COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING COMPLEMENT COMPONENT C3-ASSOCIATED DISEASES

#232
20230265424
2023-08-24

METHODS OF TREATING AND PREVENTING BACTERIAL INFECTIONS

#233
20230257740
2023-08-17

Compositions and methods for inhibiting expression of transthyretin

#234
20230235333
2023-07-27

APTAMER FOR IL-21 AND USE THEREOF

#235
20230226193
2023-07-20

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS

#236
20230212578
2023-07-06

COMPOSITIONS AND METHODS FOR TREATING HYPERTRIGLYCERIDEMIA

#237
20230203501
2023-06-29

MONOCYTE-SPECIFIC APTAMERS AND USES THEREOF FOR ENHANCING DRUG DELIVERY TO CANCER

#238
20230203498
2023-06-29

SINGLE-STRANDED OLIGONUCLEOTIDE

#239
20230203494
2023-06-29

AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME

#240
20230201363
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#241
20230201362
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#242
20230193286
2023-06-22

CYTOTOXIC T-LYMPHOCYTE BINDING APTAMERS

#243
20230193285
2023-06-22

BISPECIFIC PERSONALIZED APTAMERS

#244
20230193284
2023-06-22

TRANSMEMBRANE SERINE PROTEASE 2 (TMPRSS2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#245
20230193277
2023-06-22

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#246
20230193268
2023-06-22

APOLIPOPROTEIN E (APOE) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#247
20230192753
2023-06-22

Ribonucleic acids with 4′-thio-modified nucleotides and related methods

#248
20230174990
2023-06-08

Immunostimulatory compositions

#249
20230174981
2023-06-08

HETERONUCLEIC ACID CONTAINING MORPHOLINO NUCLEIC ACID

#250
20230172979
2023-06-08

Aptamer-Engineered Natural Killer Cells for Cell-Specific Adaptive Immunotherapy

#251
20230159933
2023-05-25

COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION

#252
20230159925
2023-05-25

ANTISENSE OLIGONUCLEOTIDE OF CALM2

#253
20230158150
2023-05-25

COMPOUND COMPRISING A NUCLEIC ACID AND A HALF-LIFE EXTENSION MOTIF

#254
20230151365
2023-05-18

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#255
20230147733
2023-05-11

OXIDIZED TUMOR CELL LYSATES ENCAPSULATED IN LIPOSOMAL SPHERICAL NUCLEIC ACIDS AS POTENT CANCER IMMUNOTHERAPEUTICS

#256
20230144623
2023-05-11

SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY

#257
20230139166
2023-05-04

RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use

#258
20230138507
2023-05-04

ALPHA-2A ADRENERGIC RECEPTOR (ADRA2A) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#259
20230136787
2023-05-04

COMPOSITIONS AND METHODS FOR SILENCING VEGF-A EXPRESSION

#260
20230133147
2023-05-04

ANGIOTENSIN-CONVERTING ENZYME 2 (ACE2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#261
20230132377
2023-04-27

OLIGONUCLEOTIDES CONJUGATES COMPRISING 7'-5'-ALPHA-ANOMERIC-BICYCLIC SUGAR NUCLEOSIDES

#262
20230126233
2023-04-27

LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#263
20230125671
2023-04-27

RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use

#264
20230122801
2023-04-20

USP10 TARGETED SELF-DELIVERABLE SIRNA COMPOSITIONS AND METHODS FOR PREVENTING OR INHIBITING FIBROSIS AND/OR SCARRING

#265
20230121944
2023-04-20

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#266
20230114649
2023-04-13

HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#267
20230110295
2023-04-13

Targeted compositions

#268
20230109020
2023-04-06

Nucleic acid and other compositions and methods for the modulation of cell membranes

#269
20230107117
2023-04-06

CONDITIONAL-siRNAS AND USES THEREOF IN TREATING CARDIAC HYPERTROPHY

#270
20230098714
2023-03-30

MICRORNA COMPOSITIONS AND METHODS OF USE

#271
20230095566
2023-03-30

ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS

#272
20230093948
2023-03-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#273
20230089915
2023-03-23

PRODUCTS AND COMPOSITIONS

#274
20230088599
2023-03-23

MIR-149-3P AND METHOD FOR TREATING METABOLIC DISEASE USING THE SAME

#275
20230068339
2023-03-02

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#276
20230064031
2023-03-02

4′-phosphate analogs and oligonucleotides comprising the same

#277
20230056569
2023-02-23

ATAXIN3 (ATXN3) RNAI AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#278
20230055931
2023-02-23

METHOD AND COMPOSITION FOR MEASUREMENT OF NITRIC OXIDE

#279
20230053332
2023-02-23

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#280
20230044994
2023-02-09

Compositions and Methods Comprising a TTR Guide RNA and a Polynucleotide Encoding an RNA-Guided DNA Binding Agent

#281
20230032974
2023-02-02

SMALL RIBOSOMAL PROTEIN SUBUNIT 25 (RPS25) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#282
20230029227
2023-01-26

Tunable Reversir™ compounds

#283
20230028937
2023-01-26

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#284
20230022185
2023-01-26

Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases

#285
20230021431
2023-01-26

Oligonucleotides for SARS-CoV-2 modulation

#286
20230002773
2023-01-05

RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use

#287
20230002772
2023-01-05

PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#288
20230002768
2023-01-05

Compositions and methods for inhibiting gene expression of alpha-1 antitrypsin

#289
20230002766
2023-01-05

CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY

#290
20220403381
2022-12-22

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#291
20220403377
2022-12-22

MODIFIED iRNA AGENTS

#292
20220401467
2022-12-22

OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF

#293
20220395580
2022-12-15

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#294
20220380774
2022-12-01

ASYMMETRIC SIRNA INHIBITING EXPRESSION OF PD-1

#295
20220380771
2022-12-01

Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof

#296
20220380762
2022-12-01

HUNTINGTIN (HTT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#297
20220372489
2022-11-24

PPM1A INHIBITORS AND METHODS OF USING SAME

#298
20220372476
2022-11-24

Dynamic pharmacokinetic-modifying anchors

#299
20220364098
2022-11-17

Compositions and methods for modulating PNPLA3 expression

#300
20220364086
2022-11-17

ANTISENSE OLIGONUCLEOTIDE CAPABLE OF ALTERING SPLICING OF DUX4 pre-mRNA