ClassID:

109221

C12N2320/30 - CPC Classification

Classification description:

Applications; Uses Special therapeutic applications

Sub-classes:
Recent Application in this class:
#1
20260158053
2026-06-11

DNA COMPOSITIONS AND RELATED METHODS

#2
20260132405
2026-05-14

Modulation of Apolipoprotein C-III (ApoCIII) Expression in Lipoprotein Lipase Deficient (LPLD) Populations

#3
20260117227
2026-04-30

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#4
20260117225
2026-04-30

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#5
20260109983
2026-04-23

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

#6
20260098260
2026-04-09

TREATING AND PREVENTING MICROBIAL INFECTIONS

#7
20260098259
2026-04-09

TREATING AND PREVENTING MICROBIAL INFECTIONS

#8
20260096999
2026-04-09

RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE

#9
20260078377
2026-03-19

CONSTRUCT COMPRISING UTR SEQUENCE THAT IMPROVES INTRACELLULAR STABILITY AND BIOSYNTHESIS OF MRNA AND USE THEREOF

#10
20260078372
2026-03-19

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL

#11
20260049310
2026-02-19

METHOD FOR REDUCING THE RISK OF A CARDIOVASCULAR EVENT WITH CONJUGATED ANTISENSE COMPOUNDS TARGETING APO(A)

#12
20260049307
2026-02-19

TREATING AND PREVENTING MICROBIAL INFECTIONS

#13
20260022392
2026-01-22

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

#14
20260009033
2026-01-08

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

#15
20260002155
2026-01-01

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#16
20260002141
2026-01-01

METHODS AND COMPOSITIONS FOR SELECTIVELY ELIMINATING CELLS OF INTEREST

#17
20260000783
2026-01-01

ANTIBODY-DRUG CONJUGATE WITH IMPROVED THERAPEUTIC WINDOW

#18
20250388897
2025-12-25

NUCLEIC ACID COMPOUNDS

#19
20250382642
2025-12-18

DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTIC APPLICATIONS

#20
20250382616
2025-12-18

SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF

#21
20250376682
2025-12-11

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN

#22
20250361509
2025-11-27

MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION

#23
20250354156
2025-11-20

Compositions and Methods for Treating Cancer

#24
20250354148
2025-11-20

DUAL-ACTING siRNA BASED MODULATION OF C9orf72

#25
20250354140
2025-11-20

CALCIUM SALTED SPHERICAL NUCLEIC ACIDS

#26
20250346906
2025-11-13

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF CD274/PD-L1 GENE

#27
20250346897
2025-11-13

COMPOSITIONS AND METHODS FOR TREATMENT OF MICROSATELLITE DNA EXPANSION DISORDERS

#28
20250340904
2025-11-06

COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY

#29
20250340890
2025-11-06

DNA APTAMERS AS UNIVERSAL INHIBITORS OF SPIKE PROTEIN/HACE2 INTERACTIONS

#30
20250333732
2025-10-30

TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS

#31
20250333730
2025-10-30

SIRNA FOR INHIBITING ANGPTL3 GENE EXPRESSION AND USE THEREOF

#32
20250332231
2025-10-30

TREATING CANCER WITH CAS ENDONUCLEASE COMPLEXES

#33
20250332187
2025-10-30

NOVEL RNA CONSTRUCT AND METHODS OF USE THEREOF FOR ENHANCING THE THERAPEUTIC EFFECTS OF CYTOTOXIC CELLS AND STEM CELLS

#34
20250313900
2025-10-09

COMPOSITIONS AND THERAPEUTIC AGENTS FOR MODULATING INFLAMMATORY RESPONSES ON BOTH TUMOR AND IMMUNE CELLS

#35
20250313843
2025-10-09

METHODS FOR TREATING HYPERCHOLESTEROLEMIA

#36
20250313836
2025-10-09

CHIRAL DESIGN

#37
20250304977
2025-10-02

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

#38
20250302983
2025-10-02

Saponin Conjugates

#39
20250283096
2025-09-11

SPHERICAL NUCLEIC ACID-BASED CONSTRUCTS AS IMMUNOSTIMULATORY AGENTS FOR PROPHYLACTIC AND THERAPEUTIC USE

#40
20250281621
2025-09-11

GPC3 APTAMERS AND VARIANTS AND USE THEREOF

#41
20250277221
2025-09-04

OLIGONUCLEOTIDES FOR PRNP MODULATION

#42
20250276060
2025-09-04

SELECTIVELY ALTERING MICROBIOTA FOR IMMUNE MODULATION

#43
20250270565
2025-08-28

SYNAPTOSOMAL MICRO RNAS AND SYNAPSE FUNCTIONS IN ALZHEIMER'S DISEASE

#44
20250250589
2025-08-07

DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTIC APPLICATIONS

#45
20250250578
2025-08-07

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

#46
20250250577
2025-08-07

ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION WITH FUNCTIONAL DOMAINS

#47
20250250562
2025-08-07

TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING

#48
20250236873
2025-07-24

Methods Of Treating Decreased Bone Mineral Density With Cluster Of Differentiation 109 (CD109) Inhibitors

#49
20250236869
2025-07-24

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#50
20250213724
2025-07-03

RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES

#51
20250207136
2025-06-26

Use of Telomerase Inhibitors for the Treatment of Myeloproliferative Disorders and Myeloproliferative Neoplasms

#52
20250197856
2025-06-19

METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY

#53
20250188473
2025-06-12

Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors

#54
20250179495
2025-06-05

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

#55
20250163420
2025-05-22

Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128

#56
20250163414
2025-05-22

ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF

#57
20250154507
2025-05-15

MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD

#58
20250154480
2025-05-15

TREATMENT FOR NUCLEOTIDE REPEAT EXPANSION DISEASE

#59
20250145991
2025-05-08

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#60
20250145952
2025-05-08

T CELLS WITH IMPROVED FUNCTIONALITY

#61
20250136980
2025-05-01

MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOPATHIES

#62
20250115912
2025-04-10

METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS

#63
20250101434
2025-03-27

Interferon Production Using Short RNA Duplexes

#64
20250092402
2025-03-20

MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER

#65
20250084435
2025-03-13

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#66
20250082735
2025-03-13

PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES

#67
20250075211
2025-03-06

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES

#68
20250075208
2025-03-06

OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION

#69
20250066792
2025-02-27

COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEIN KINASE (DMPK) EXPRESSION

#70
20250066786
2025-02-27

ANGELMAN SYNDROME ANTISENSE TREATMENT

#71
20250043286
2025-02-06

METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE

#72
20250043284
2025-02-06

OLIGONUCLEOTIDES FOR SNCA MODULATION

#73
20250034566
2025-01-30

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#74
20250019763
2025-01-16

HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS

#75
20250019719
2025-01-16

Purification and Purity Assessment of RNA Molecules Synthesized with Modified Nucleosides

#76
20250011784
2025-01-09

RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS

#77
20250003969
2025-01-02

METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESISTANT INFLAMMATORY DISEASES

#78
20250000889
2025-01-02

METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS

#79
20240417721
2024-12-19

SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES

#80
20240417706
2024-12-19

SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

#81
20240409941
2024-12-12

BIOACTIVE RENAL CELLS

#82
20240409929
2024-12-12

TRANSTHYRETIN (TTR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#83
20240401063
2024-12-05

Aptamer for DKK1 and Use Thereof

#84
20240401060
2024-12-05

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#85
20240398848
2024-12-05

MLK-Regulated microRNAs in Angiogenesis and Tumor Development

#86
20240376478
2024-11-14

Antisense Oligonucleotide (ASO) Gene Inhibition and Treatment

#87
20240368248
2024-11-07

GROWTH FACTOR ANTAGONISTS FOR ORGAN TRANSPLANT ALLOIMMUNITY AND ARTERIOSCLEROSIS

#88
20240360447
2024-10-31

COMPOUNDS TARGETING PMP22 FOR THE TREATMENT OF CHARCOT-MARIE-TOOTH DISEASE

#89
20240352120
2024-10-24

COSTIMULATORY B7-H1 IN RENAL CELL CARCINOMA PATIENTS: INDICATOR OF TUMOR AGGRESSIVENESS AND POTENTIAL THERAPEUTIC TARGET

#90
20240336919
2024-10-10

RNA EDITING

#91
20240327844
2024-10-03

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

#92
20240325427
2024-10-03

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#93
20240318201
2024-09-26

RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DUX4

#94
20240316206
2024-09-26

NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS

#95
20240309387
2024-09-19

TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#96
20240309386
2024-09-19

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE

#97
20240309379
2024-09-19

CTLA-4 APTAMER CONJUGATES

#98
20240301510
2024-09-12

ASSESSING RISK FOR COLORECTAL ADENOMA RECURRENCE BY NONINVASIVE MEANS

#99
20240301424
2024-09-12

MANIPULATED IMMUNOREGULATORY ELEMENT AND IMMUNITY ALTERED THEREBY

#100
20240301412
2024-09-12

COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION

#101
20240294916
2024-09-05

SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF

#102
20240279661
2024-08-22

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

#103
20240279652
2024-08-22

RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES

#104
20240271136
2024-08-15

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#105
20240254486
2024-08-01

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#106
20240240202
2024-07-18

COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY

#107
20240240184
2024-07-18

MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION

#108
20240240183
2024-07-18

Heteronucleic acid containing scpBNA or AmNA

#109
20240229045
2024-07-11

Aptamer for specifically recognizing soluble ST2 protein and application of the same

#110
20240209359
2024-06-27

METHODS, SYSTEMS, AND APPARATUS FOR IDENTIFYING TARGET SEQUENCES FOR CAS ENZYMES OR CRISPR-CAS SYSTEMS FOR TARGET SEQUENCES AND CONVEYING RESULTS THEREOF

#111
20240200079
2024-06-20

Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors

#112
20240191235
2024-06-13

TREATMENT OF TUMORS WITH MIRNA TARGETING CDK4/CDK6

#113
20240191231
2024-06-13

SPINAL MUSCULAR ATROPHY (SMA) TREATMENT VIA TARGETING OF SMN2 SPLICE SITE INHIBITORY SEQUENCES

#114
20240175033
2024-05-30

TMEM173 saRNA Compositions and Methods of Use

#115
20240175014
2024-05-30

MATERIALS AND METHODS FOR TREATMENT OF ALPHA-1 ANTITRYPSIN DEFICIENCY

#116
20240175013
2024-05-30

BIALLELIC KNOCKOUT OF TRAC

#117
20240165267
2024-05-23

MODIFIED NUCLEIC ACID MOLECULES AND USES THEREOF

#118
20240158955
2024-05-16

OLIGONUCLEIC ACID VARIANT LIBRARIES AND SYNTHESIS THEREOF

#119
20240148875
2024-05-09

Lipid formulations for delivery of therapeutic agents

#120
20240141360
2024-05-02

MODULATORS AND MODULATION OF THE RECEPTOR FOR ADVANCED GLYCATION END-PRODUCTS RNA

#121
20240141355
2024-05-02

MODULATION OF GYS1 EXPRESSION

#122
20240139294
2024-05-02

METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION

#123
20240138418
2024-05-02

METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS

#124
20240132892
2024-04-25

OLIGONUCLEOTIDE-BASED MODULATION OF C9orf72

#125
20240132885
2024-04-25

MODULATION OF TRANSTHYRETIN EXPRESSION

#126
20240131050
2024-04-25

INHIBITION OF EXPANSION AND FUNCTION OF PATHOGENIC AGE-ASSOCIATED B CELLS AND USE FOR THE PREVENTION AND TREATMENT OF AUTOIMMUNE DISEASE

#127
20240124882
2024-04-18

PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#128
20240117432
2024-04-11

METHODS AND KITS FOR DETECTING A RISK FOR DEVELOPING NEUROLOGICAL OR NEUROPHYSIOLOGICAL DISORDERS

#129
20240102107
2024-03-28

METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY

#130
20240102010
2024-03-28

Novel Structurally Designed shRNAs

#131
20240100166
2024-03-28

NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS

#132
20240093194
2024-03-21

MIR-7-5P MIMIC FOR INHIBITING MIGRATION AND INVASION OF BREAST CANCER, SCREENING METHOD AND APPLICATION THEREOF

#133
20240084306
2024-03-14

LOCALIZED THERAPY OF LOWER AIRWAYS INFLAMMATORY DISORDERS WITH PROINFLAMMATORY CYTOKINE INHIBITORS

#134
20240035035
2024-02-01

COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING VIRAL INFECTIONS

#135
20240035032
2024-02-01

Oligomers and oligomer conjugates

#136
20240026355
2024-01-25

COMPOSITIONS FOR AND METHODS OF ENHANCING TISSUE REGENERATION

#137
20240018517
2024-01-18

MODULATING HEMATAOPOIESIS AND MYLEOID CELL PRODUCTION

#138
20240018486
2024-01-18

RNA PREPARATIONS COMPRISING PURIFIED MODIFIED RNA FOR REPROGRAMMING CELLS

#139
20240002854
2024-01-04

Albumin Production and Cell Proliferation

#140
20230392151
2023-12-07

NUCLEIC ACID MOLECULES WITH INCREASED GENE SILENCING ACTIVITY AND USES THEREOF

#141
20230365965
2023-11-16

SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#142
20230364123
2023-11-16

Methods for treating or preventing ophthalmological conditions

#143
20230364122
2023-11-16

METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS

#144
20230357763
2023-11-09

Morpholinos with Increased Delivery Efficiency

#145
20230340486
2023-10-26

IN UTERO AND POSTNATAL GENE EDITING AND THERAPY FOR TREATMENT OF MONOGENIC DISEASES, INCLUDING MUCOPOLYSACCHARIDOSIS TYPE 1H AND OTHER DISORDERS

#146
20230340483
2023-10-26

DOUBLE-STRANDED RNA THAT INHIBITS PRODUCTION OF HEPATITIS B VIRUS PROTEIN AND PHARMACEUTICAL COMPOSITION

#147
20230340473
2023-10-26

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#148
20230332158
2023-10-19

NOVEL USE OF HIC-5 INHIBITOR

#149
20230332152
2023-10-19

Angelman syndrome antisense treatment

#150
20230323388
2023-10-12

Treatment of amyotrophic lateral sclerosis (ALS)

#151
20230323356
2023-10-12

METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS

#152
20230313229
2023-10-05

Genetic Construct

#153
20230313203
2023-10-05

FLUOROARABINO NUCLEIC ACID (FANA) APTAMERS THAT BIND SARS-2 RECEPTOR BINDING DOMAIN AND BLOCK BINDING TO THE ACE2 CELLULAR RECEPTOR

#154
20230310402
2023-10-05

CORNEAL ENDOTHELIUM ECM THERAPEUTIC MEDICAMENTS

#155
20230304003
2023-09-28

EXPRESSION CONTROL USING A REGULATABLE INTRON

#156
20230287411
2023-09-14

METHODS FOR ENGINEERING NON-NEURONAL CELLS INTO NEURONS AND USING NEWLY ENGINEERED NEURONS TO TREAT NEURODEGENERATIVE DISEASES

#157
20230285538
2023-09-14

EFFICACIOUS MRNA VACCINES

#158
20230279393
2023-09-07

Treatment of Airway Conditions by Modulation of MiR200 Family MicroRNAs

#159
20230279392
2023-09-07

Single-stranded RNA-editing oligonucleotides

#160
20230272388
2023-08-31

MIR-96-5P INHIBITOR AND PHARMACEUTICAL COMPOSITION CONTAINING SAME

#161
20230265049
2023-08-24

Lipidoids for Nucleic Acid Transfection and Use Thereof

#162
20230257740
2023-08-17

Compositions and methods for inhibiting expression of transthyretin

#163
20230255999
2023-08-17

DNA compositions and related methods

#164
20230250431
2023-08-10

RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE

#165
20230250427
2023-08-10

NUTRITIONAL COMPOSITION COMPRISING MIR-3126

#166
20230250408
2023-08-10

NOVEL HYALURONIDASE VARIANTS WITH IMPROVED STABILITY AND PHARMACEUTICAL COMPOSITION COMPRISING THE SAME

#167
20230250398
2023-08-10

PROCESS FOR PRODUCING LIVER CELLS

#168
20230248831
2023-08-10

Lipid formulations for delivery of therapeutic agents

#169
20230248822
2023-08-10

Selectively altering microbiota for immune modulation

#170
20230248768
2023-08-10

ENGINEERED IMMUNE CELL FOR ALLOTRANSPLANTATION

#171
20230242913
2023-08-03

STING-DEPENDENT ACTIVATORS FOR TREATMENT OF DISEASE

#172
20230235331
2023-07-27

COMPOUNDS AND METHODS FOR REDUCING MSH3 EXPRESSION

#173
20230235323
2023-07-27

Compounds and Methods for Reducing ATXN3 Expression

#174
20230220403
2023-07-13

SPECIFIC DECOLONIZATION OF ANTIBIOTIC RESISTANT BACTERIA FOR PROPHYLACTIC PURPOSES

#175
20230220385
2023-07-13

MICRORNA AS A THERAPEUTIC AGENT

#176
20230212540
2023-07-06

Gene editing systems comprising an RNA guide targeting lactate dehydrogenase a (LDHA) and uses thereof

#177
20230212514
2023-07-06

MONOCYTE PURIFICATION METHOD IN PERIPHERAL BLOOD RAW MATERIAL COLLECTION/ FREEZING-THAWING STEP

#178
20230203497
2023-06-29

DYNAMIN 2 INHIBITOR FOR THE TREATMENT OF CENTRONUCLEAR MYOPATHIES

#179
20230203495
2023-06-29

FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE SKIN GRAFT HEALING

#180
20230201317
2023-06-29

PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES

#181
20230193257
2023-06-22

TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING

#182
20230192879
2023-06-22

METHODS FOR THE DIAGNOSIS AND TREATMENT OF CYTOKINE RELEASE SYNDROME

#183
20230183704
2023-06-15

Use of Telomerase Inhibitors for the Treatment of Myeloproliferative Disorders and Myeloproliferative Neoplasms

#184
20230181698
2023-06-15

METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION

#185
20230181651
2023-06-15

TREATMENT OF VIRUS-INDUCED ACUTE RESPIRATORY DISTRESS SYNDROME

#186
20230181528
2023-06-15

COMPOSITIONS AND METHODS FOR TREATING NEOPLASIA

#187
20230174982
2023-06-08

ENGINEERED NUCLEIC ACIDS AND USES THEREOF

#188
20230167440
2023-06-01

METHOD OF STIMULATING PROLIFERATION OF A CELL

#189
20230159925
2023-05-25

ANTISENSE OLIGONUCLEOTIDE OF CALM2

#190
20230158150
2023-05-25

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RNA FOR TREATMENT OR PROPHYLAXIS OF A LIVER DISEASE

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ONCOLYTIC VIRAL VECTORS AND USES THEREOF

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Angleman syndrome antisense treatment

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COMPOSITIONS AND METHODS TO TREAT NEUROLOGICAL DISEASES

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RNAS FOR COMPLEMENT INHIBITION

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Thrombin Binding Circular Aptamer and Use Thereof

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ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF CANCER STEM CELLS

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Modulation of Angiopoietin-Like 3 Expression

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RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS

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IMPROVED ANTIBODY-OLIGONUCLEOTIDE CONJUGATE

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SEQUENCE-SPECIFIC IN VIVO CELL TARGETING

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RNA-Editing Enzyme-Recruiting Oligonucleotides and Uses Thereof

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HUMAN HEAD AND NECK CANCER TREATMENT

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miRNAS FOR REDUCING VENTRICLE ENLARGEMENT

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CONJUGATES AND METHODS FOR TREATING ACROMEGALY

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METHOD OF MODULATING ADIPOSITY

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TREATING AND PREVENTING MICROBIAL INFECTIONS

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RNA INTERFERENCE-INDUCING NUCLEIC ACID INHIBITING NONCANONICAL TARGETS OF MICRO RNA, AND USE FOR SAME

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Treating and preventing microbial infections

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OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA

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APTAMERS AGAINST GLIOBLASTOMA

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Treatment of amyotrophic lateral sclerosis (ALS)

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SIRT1-SARNA COMPOSITIONS AND METHODS OF USE

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Nanoparticle to target cancer

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MOLECULAR MARKER DETECTION AND REGULATING METHODS IN DE-SERVITIZATION STATE OF CELLS

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OLIGOMERS

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NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL

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Novel Process for Preparing Rhenium Chelated MAG3 Oligonucleotides

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VIRAL VECTORS FOR THE TREATMENT OF DIABETES

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CD40 Specific DNA Aptamers as Vaccine Adjuvants

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T-lymphocyte binding aptamers

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MicroRNA-198 as a tumor suppressor in ovarian cancer

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Methods for treating or preventing ophthalmological conditions

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Nucleic acids for inhibiting expression of LPA in a cell

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NOVEL METHOD FOR MONITORING ENDOMETRIOSIS AND ASSOCIATED DISORDERS

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RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS

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COMPOSITIONS COMPRISING ALTERNATING 2'-MODIFIED NUCLEOSIDES FOR USE IN GENE MODULATION

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Mammalian somatic cell with modified RNA encoding reprogramming factors

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Methods to identify and treat subjects having corticosteroid-resistant inflammatory diseases

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COMPOSITIONS AND METHODS FOR IN VIVO EXCISION OF HIV-1 PROVIRAL DNA

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NOVEL NUCLEIC ACID MOLECULES AND THEIR USE IN THERAPY

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CHMP2A as a Regulator of Natural Killer Cell-Mediated Activity

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CAS9 VARIANTS WITH ENHANCED SPECIFICITY

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CTLA-4 aptamer conjugates

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NEW BIOMARKERS AND BIOTARGETS IN RENAL CELL CARCINOMA

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COMPOSITIONS FOR SUPPRESSING TRIM28 AND USES THEREOF

#291
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TARGETING SENESCENT CELLS

#292
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DIAGNOSIS AND TREATMENT OF MEDULLOBLASTOMA

#293
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NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL

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Peptides and combination of peptides for use in immunotherapy against ovarian cancer and other cancers

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COMPOSITIONS AND METHODS FOR ALLEVIATING PAIN

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COMPOSITION COMPRISING A MIXTURE OF DNA MOLECULES, USES THEREOF AS BIOLOGICAL INHIBITOR AND METHOD FOR PRODUCTION

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Polycomb-associated Non-Coding RNAs

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Therapeutic alteration of transplantable tissues through or exposure to RNA interference molecules

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EXOSOMES AND MICRO-RIBONUCLEIC ACIDS FOR TISSUE REGENERATION

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ADVANCED CHIMERIC ANTIGEN RECEPTOR VECTORS FOR TARGETING SOLID TUMORS