109221 ⎘
Applications; Uses Special therapeutic applications
Sub-classes:DNA COMPOSITIONS AND RELATED METHODS
#2Modulation of Apolipoprotein C-III (ApoCIII) Expression in Lipoprotein Lipase Deficient (LPLD) Populations
#3COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#4COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#5HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#6TREATING AND PREVENTING MICROBIAL INFECTIONS
#7TREATING AND PREVENTING MICROBIAL INFECTIONS
#8RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE
#9CONSTRUCT COMPRISING UTR SEQUENCE THAT IMPROVES INTRACELLULAR STABILITY AND BIOSYNTHESIS OF MRNA AND USE THEREOF
#10NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#11METHOD FOR REDUCING THE RISK OF A CARDIOVASCULAR EVENT WITH CONJUGATED ANTISENSE COMPOUNDS TARGETING APO(A)
#12TREATING AND PREVENTING MICROBIAL INFECTIONS
#13CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#14ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#15SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#16METHODS AND COMPOSITIONS FOR SELECTIVELY ELIMINATING CELLS OF INTEREST
#17ANTIBODY-DRUG CONJUGATE WITH IMPROVED THERAPEUTIC WINDOW
#18NUCLEIC ACID COMPOUNDS
#19DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTIC APPLICATIONS
#20SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#21COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
#22MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#23Compositions and Methods for Treating Cancer
#24DUAL-ACTING siRNA BASED MODULATION OF C9orf72
#25CALCIUM SALTED SPHERICAL NUCLEIC ACIDS
#26COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF CD274/PD-L1 GENE
#27COMPOSITIONS AND METHODS FOR TREATMENT OF MICROSATELLITE DNA EXPANSION DISORDERS
#28COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#29DNA APTAMERS AS UNIVERSAL INHIBITORS OF SPIKE PROTEIN/HACE2 INTERACTIONS
#30TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#31SIRNA FOR INHIBITING ANGPTL3 GENE EXPRESSION AND USE THEREOF
#32TREATING CANCER WITH CAS ENDONUCLEASE COMPLEXES
#33NOVEL RNA CONSTRUCT AND METHODS OF USE THEREOF FOR ENHANCING THE THERAPEUTIC EFFECTS OF CYTOTOXIC CELLS AND STEM CELLS
#34COMPOSITIONS AND THERAPEUTIC AGENTS FOR MODULATING INFLAMMATORY RESPONSES ON BOTH TUMOR AND IMMUNE CELLS
#35METHODS FOR TREATING HYPERCHOLESTEROLEMIA
#36CHIRAL DESIGN
#37CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#38Saponin Conjugates
#39SPHERICAL NUCLEIC ACID-BASED CONSTRUCTS AS IMMUNOSTIMULATORY AGENTS FOR PROPHYLACTIC AND THERAPEUTIC USE
#40GPC3 APTAMERS AND VARIANTS AND USE THEREOF
#41OLIGONUCLEOTIDES FOR PRNP MODULATION
#42SELECTIVELY ALTERING MICROBIOTA FOR IMMUNE MODULATION
#43SYNAPTOSOMAL MICRO RNAS AND SYNAPSE FUNCTIONS IN ALZHEIMER'S DISEASE
#44DELIVERY, ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTIC APPLICATIONS
#45CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#46ENGINEERING AND OPTIMIZATION OF SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION WITH FUNCTIONAL DOMAINS
#47TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING
#48Methods Of Treating Decreased Bone Mineral Density With Cluster Of Differentiation 109 (CD109) Inhibitors
#49EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#50RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES
#51Use of Telomerase Inhibitors for the Treatment of Myeloproliferative Disorders and Myeloproliferative Neoplasms
#52METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#53Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors
#54ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#55Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#56ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF
#57MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
#58TREATMENT FOR NUCLEOTIDE REPEAT EXPANSION DISEASE
#59EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#60T CELLS WITH IMPROVED FUNCTIONALITY
#61MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOPATHIES
#62METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS
#63Interferon Production Using Short RNA Duplexes
#64MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER
#65TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#66PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES
#67TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES
#68OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION
#69COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEIN KINASE (DMPK) EXPRESSION
#70ANGELMAN SYNDROME ANTISENSE TREATMENT
#71METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#72OLIGONUCLEOTIDES FOR SNCA MODULATION
#73COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#74HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS
#75Purification and Purity Assessment of RNA Molecules Synthesized with Modified Nucleosides
#76RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS
#77METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESISTANT INFLAMMATORY DISEASES
#78METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS
#79SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
#80SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#81BIOACTIVE RENAL CELLS
#82TRANSTHYRETIN (TTR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#83Aptamer for DKK1 and Use Thereof
#84COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#85MLK-Regulated microRNAs in Angiogenesis and Tumor Development
#86Antisense Oligonucleotide (ASO) Gene Inhibition and Treatment
#87GROWTH FACTOR ANTAGONISTS FOR ORGAN TRANSPLANT ALLOIMMUNITY AND ARTERIOSCLEROSIS
#88COMPOUNDS TARGETING PMP22 FOR THE TREATMENT OF CHARCOT-MARIE-TOOTH DISEASE
#89COSTIMULATORY B7-H1 IN RENAL CELL CARCINOMA PATIENTS: INDICATOR OF TUMOR AGGRESSIVENESS AND POTENTIAL THERAPEUTIC TARGET
#90RNA EDITING
#91ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#92TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#93RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DUX4
#94NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#95TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#96COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#97CTLA-4 APTAMER CONJUGATES
#98ASSESSING RISK FOR COLORECTAL ADENOMA RECURRENCE BY NONINVASIVE MEANS
#99MANIPULATED IMMUNOREGULATORY ELEMENT AND IMMUNITY ALTERED THEREBY
#100COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION
#101SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#102HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#103RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#104COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#105COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#106COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#107MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#108Heteronucleic acid containing scpBNA or AmNA
#109Aptamer for specifically recognizing soluble ST2 protein and application of the same
#110METHODS, SYSTEMS, AND APPARATUS FOR IDENTIFYING TARGET SEQUENCES FOR CAS ENZYMES OR CRISPR-CAS SYSTEMS FOR TARGET SEQUENCES AND CONVEYING RESULTS THEREOF
#111Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors
#112TREATMENT OF TUMORS WITH MIRNA TARGETING CDK4/CDK6
#113SPINAL MUSCULAR ATROPHY (SMA) TREATMENT VIA TARGETING OF SMN2 SPLICE SITE INHIBITORY SEQUENCES
#114TMEM173 saRNA Compositions and Methods of Use
#115MATERIALS AND METHODS FOR TREATMENT OF ALPHA-1 ANTITRYPSIN DEFICIENCY
#116BIALLELIC KNOCKOUT OF TRAC
#117MODIFIED NUCLEIC ACID MOLECULES AND USES THEREOF
#118OLIGONUCLEIC ACID VARIANT LIBRARIES AND SYNTHESIS THEREOF
#119Lipid formulations for delivery of therapeutic agents
#120MODULATORS AND MODULATION OF THE RECEPTOR FOR ADVANCED GLYCATION END-PRODUCTS RNA
#121MODULATION OF GYS1 EXPRESSION
#122METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#123METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS
#124OLIGONUCLEOTIDE-BASED MODULATION OF C9orf72
#125MODULATION OF TRANSTHYRETIN EXPRESSION
#126INHIBITION OF EXPANSION AND FUNCTION OF PATHOGENIC AGE-ASSOCIATED B CELLS AND USE FOR THE PREVENTION AND TREATMENT OF AUTOIMMUNE DISEASE
#127PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#128METHODS AND KITS FOR DETECTING A RISK FOR DEVELOPING NEUROLOGICAL OR NEUROPHYSIOLOGICAL DISORDERS
#129METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY
#130Novel Structurally Designed shRNAs
#131NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#132MIR-7-5P MIMIC FOR INHIBITING MIGRATION AND INVASION OF BREAST CANCER, SCREENING METHOD AND APPLICATION THEREOF
#133LOCALIZED THERAPY OF LOWER AIRWAYS INFLAMMATORY DISORDERS WITH PROINFLAMMATORY CYTOKINE INHIBITORS
#134COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING VIRAL INFECTIONS
#135Oligomers and oligomer conjugates
#136COMPOSITIONS FOR AND METHODS OF ENHANCING TISSUE REGENERATION
#137MODULATING HEMATAOPOIESIS AND MYLEOID CELL PRODUCTION
#138RNA PREPARATIONS COMPRISING PURIFIED MODIFIED RNA FOR REPROGRAMMING CELLS
#139Albumin Production and Cell Proliferation
#140NUCLEIC ACID MOLECULES WITH INCREASED GENE SILENCING ACTIVITY AND USES THEREOF
#141SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#142Methods for treating or preventing ophthalmological conditions
#143METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS
#144Morpholinos with Increased Delivery Efficiency
#145IN UTERO AND POSTNATAL GENE EDITING AND THERAPY FOR TREATMENT OF MONOGENIC DISEASES, INCLUDING MUCOPOLYSACCHARIDOSIS TYPE 1H AND OTHER DISORDERS
#146DOUBLE-STRANDED RNA THAT INHIBITS PRODUCTION OF HEPATITIS B VIRUS PROTEIN AND PHARMACEUTICAL COMPOSITION
#147SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#148NOVEL USE OF HIC-5 INHIBITOR
#149Angelman syndrome antisense treatment
#150Treatment of amyotrophic lateral sclerosis (ALS)
#151METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS
#152Genetic Construct
#153FLUOROARABINO NUCLEIC ACID (FANA) APTAMERS THAT BIND SARS-2 RECEPTOR BINDING DOMAIN AND BLOCK BINDING TO THE ACE2 CELLULAR RECEPTOR
#154CORNEAL ENDOTHELIUM ECM THERAPEUTIC MEDICAMENTS
#155EXPRESSION CONTROL USING A REGULATABLE INTRON
#156METHODS FOR ENGINEERING NON-NEURONAL CELLS INTO NEURONS AND USING NEWLY ENGINEERED NEURONS TO TREAT NEURODEGENERATIVE DISEASES
#157EFFICACIOUS MRNA VACCINES
#158Treatment of Airway Conditions by Modulation of MiR200 Family MicroRNAs
#159Single-stranded RNA-editing oligonucleotides
#160MIR-96-5P INHIBITOR AND PHARMACEUTICAL COMPOSITION CONTAINING SAME
#161Lipidoids for Nucleic Acid Transfection and Use Thereof
#162Compositions and methods for inhibiting expression of transthyretin
#163DNA compositions and related methods
#164RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE
#165NUTRITIONAL COMPOSITION COMPRISING MIR-3126
#166NOVEL HYALURONIDASE VARIANTS WITH IMPROVED STABILITY AND PHARMACEUTICAL COMPOSITION COMPRISING THE SAME
#167PROCESS FOR PRODUCING LIVER CELLS
#168Lipid formulations for delivery of therapeutic agents
#169Selectively altering microbiota for immune modulation
#170ENGINEERED IMMUNE CELL FOR ALLOTRANSPLANTATION
#171STING-DEPENDENT ACTIVATORS FOR TREATMENT OF DISEASE
#172COMPOUNDS AND METHODS FOR REDUCING MSH3 EXPRESSION
#173Compounds and Methods for Reducing ATXN3 Expression
#174SPECIFIC DECOLONIZATION OF ANTIBIOTIC RESISTANT BACTERIA FOR PROPHYLACTIC PURPOSES
#175MICRORNA AS A THERAPEUTIC AGENT
#176Gene editing systems comprising an RNA guide targeting lactate dehydrogenase a (LDHA) and uses thereof
#177MONOCYTE PURIFICATION METHOD IN PERIPHERAL BLOOD RAW MATERIAL COLLECTION/ FREEZING-THAWING STEP
#178DYNAMIN 2 INHIBITOR FOR THE TREATMENT OF CENTRONUCLEAR MYOPATHIES
#179FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE SKIN GRAFT HEALING
#180PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES
#181TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING
#182METHODS FOR THE DIAGNOSIS AND TREATMENT OF CYTOKINE RELEASE SYNDROME
#183Use of Telomerase Inhibitors for the Treatment of Myeloproliferative Disorders and Myeloproliferative Neoplasms
#184METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#185TREATMENT OF VIRUS-INDUCED ACUTE RESPIRATORY DISTRESS SYNDROME
#186COMPOSITIONS AND METHODS FOR TREATING NEOPLASIA
#187ENGINEERED NUCLEIC ACIDS AND USES THEREOF
#188METHOD OF STIMULATING PROLIFERATION OF A CELL
#189ANTISENSE OLIGONUCLEOTIDE OF CALM2
#190COMPOUND COMPRISING A NUCLEIC ACID AND A HALF-LIFE EXTENSION MOTIF
#191RNA FOR TREATMENT OR PROPHYLAXIS OF A LIVER DISEASE
#192MODIFIED SHORT-INTERFERING RNA COMPOSITIONS AND THEIR USE IN THE TREATMENT OF CANCER
#193ALPHA-2A ADRENERGIC RECEPTOR (ADRA2A) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#194MANNAN BINDING LECTIN SERINE PEPTIDASE 2 (MASP2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#195ONCOLYTIC VIRAL VECTORS AND USES THEREOF
#196Angleman syndrome antisense treatment
#197Transthyretin (TTR) iRNA compositions and methods of use thereof
#198COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-1 ANTITRYPSIN EXPRESSION
#199COMPOSITIONS AND METHODS TO TREAT NEUROLOGICAL DISEASES
#200RNAS FOR COMPLEMENT INHIBITION
#201Modulation Of Endoplasmic Reticulum Aminopeptidase 2 (ERAP2)-Mediated Immune Response
#202INHIBITION OF TAP63 REGULATED ONCOGENIC LONG NON-CODING RNAS (TROLLS) IN THE TREATMENT OF CANCER
#203Thrombin Binding Circular Aptamer and Use Thereof
#204Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors
#205COMPOUNDS AND METHODS FOR REDUCING APP EXPRESSION
#206COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#207ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF CANCER STEM CELLS
#208Compositions and methods for treating cancer
#209Nucleic acids for inhibiting expression of C3 in a cell
#210Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#211Nucleic acids for inhibiting expression of PROS1 in a cell
#212Modulators and modulation of the receptor for advanced glycation end-products RNA
#213RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#214CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY
#215Hippo and dystrophin complex signaling in cardiomyocyte renewal
#216COMPOSITIONS AND METHODS FOR DECREASING TAU EXPRESSION
#217METHODS OF TREATING DEMENTIA ASSOCIATED WITH ALZHEIMER'S DISEASE WITH PROTECTIVE PROTEIN/CATHEPSIN A (PPCA)
#218Modulation of Angiopoietin-Like 3 Expression
#219COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#220COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#221COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF
#222RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS
#223HUNTINGTIN (HTT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#224Inhibitors Of RNA Editing And Uses Thereof
#225Methods of treating liver diseases with phosphodiesterase 3B (PDE3B) inhibitors
#226RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#227Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#228METHOD OF STIMULATING PROLIFERATION OF A CELL
#229ANTISENSE OLIGONUCLEOTIDES (ASOs) DESIGNED TO INHIBIT IMMUNE CHECKPOINT PROTEINS
#230COMPOSITION FOR DIAGNOSIS OR TREATMENT OF A CONDITION ASSOCIATED WITH INCREASED ACTIVITY OF EIF4E COMPRISING AN EIF4E INHIBITOR
#231Oligonucleotide-ligand conjugates and process for their preparation
#232Methods for treating SARS-CoV-2 infection
#233Nucleic Acid Compounds that Bind to Retinoic Acid-Inducible Gene I Protein
#234NUCLEIC ACID THAT INHIBITS EXPRESSION OF MEX3B GENE, MEX3B GENE EXPRESSION INHIBITING AGENT, METHOD FOR INHIBITING MEX3B GENE EXPRESSION, AND PROPHYLACTIC OR THERAPEUTIC AGENT FOR DISEASE CAUSED BY MEX3B GENE EXPRESSION
#235VASCULOGENIC FIBROBLASTS
#236SMALL INTERFERING RNA (siRNA) FOR INHIBITING THE EXPRESSION OF MINI-CHROMOSOME MAINTENANCE 7 (MCM7) GENE, AND COMPOSITION AND USE THEREOF
#237COMPOSITIONS, SYSTEMS AND METHODS FOR CELL THERAPY
#238IMPROVED ANTIBODY-OLIGONUCLEOTIDE CONJUGATE
#239SEQUENCE-SPECIFIC IN VIVO CELL TARGETING
#240METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#241RNA-Editing Enzyme-Recruiting Oligonucleotides and Uses Thereof
#242PROCESS OF DELIVERING SMALL RNAS TO SPERM
#243Strategy to increase anti-viral, anti-microbial, and anti-fungal defense
#244HUMAN HEAD AND NECK CANCER TREATMENT
#245miRNAS FOR REDUCING VENTRICLE ENLARGEMENT
#246A Method Of Promoting Survival And/Or Function Of A Motor Neuron And Related Agents, Uses And Methods
#247COMPOSITIONS AND METHODS FOR MODULATING SPLICING AND PROTEIN EXPRESSION
#248Methods to detect motor neuron disease comprising micro-RNAs
#249Treating and preventing microbial infections
#250CONJUGATES AND METHODS FOR TREATING ACROMEGALY
#251METHOD OF MODULATING ADIPOSITY
#252TREATING AND PREVENTING MICROBIAL INFECTIONS
#253COMPOSITIONS AND METHODS FOR MATURING STEM CELL-DERIVED BETA CELLS
#254RNA INTERFERENCE-INDUCING NUCLEIC ACID INHIBITING NONCANONICAL TARGETS OF MICRO RNA, AND USE FOR SAME
#255HSD17B13 variants and uses thereof
#256Treating and preventing microbial infections
#257COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#258OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA
#259Compositions and Methods for Monitoring, Diagnosis, Detection and Treatment of Cancer
#260APTAMERS AGAINST GLIOBLASTOMA
#261Compositions and methods for monitoring, diagnosis, prognosis, detection, and treatment of cancer
#262MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#263CORRECTION OF THE TWO MOST PREVALENT USH2A MUTATIONS BY GENOME EDITING
#264MODULATION OF APOLIPOPROTEIN C-III (APOCIII) EXPRESSION IN LIPOPROTEIN LIPASE DEFICIENT (LPLD) POPULATIONS
#265Treatment of amyotrophic lateral sclerosis (ALS)
#266SIRT1-SARNA COMPOSITIONS AND METHODS OF USE
#267Nanoparticle to target cancer
#268RNAi agents for inhibiting expression of HIF-2 alpha (), compositions thereof, and methods of use
#269MOLECULAR MARKER DETECTION AND REGULATING METHODS IN DE-SERVITIZATION STATE OF CELLS
#270OLIGOMERS
#271NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL
#272Novel Process for Preparing Rhenium Chelated MAG3 Oligonucleotides
#273VIRAL VECTORS FOR THE TREATMENT OF DIABETES
#274CD40 Specific DNA Aptamers as Vaccine Adjuvants
#275T-lymphocyte binding aptamers
#276MicroRNA-198 as a tumor suppressor in ovarian cancer
#277Methods for treating or preventing ophthalmological conditions
#278Nucleic acids for inhibiting expression of LPA in a cell
#279NOVEL METHOD FOR MONITORING ENDOMETRIOSIS AND ASSOCIATED DISORDERS
#280RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#281COMPOSITIONS COMPRISING ALTERNATING 2'-MODIFIED NUCLEOSIDES FOR USE IN GENE MODULATION
#282Mammalian somatic cell with modified RNA encoding reprogramming factors
#283Methods to identify and treat subjects having corticosteroid-resistant inflammatory diseases
#284COMPOSITIONS AND METHODS FOR IN VIVO EXCISION OF HIV-1 PROVIRAL DNA
#285NOVEL NUCLEIC ACID MOLECULES AND THEIR USE IN THERAPY
#286CHMP2A as a Regulator of Natural Killer Cell-Mediated Activity
#287CAS9 VARIANTS WITH ENHANCED SPECIFICITY
#288CTLA-4 aptamer conjugates
#289NEW BIOMARKERS AND BIOTARGETS IN RENAL CELL CARCINOMA
#290COMPOSITIONS FOR SUPPRESSING TRIM28 AND USES THEREOF
#291TARGETING SENESCENT CELLS
#292DIAGNOSIS AND TREATMENT OF MEDULLOBLASTOMA
#293NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#294Peptides and combination of peptides for use in immunotherapy against ovarian cancer and other cancers
#295COMPOSITIONS AND METHODS FOR ALLEVIATING PAIN
#296COMPOSITION COMPRISING A MIXTURE OF DNA MOLECULES, USES THEREOF AS BIOLOGICAL INHIBITOR AND METHOD FOR PRODUCTION
#297Polycomb-associated Non-Coding RNAs
#298Therapeutic alteration of transplantable tissues through or exposure to RNA interference molecules
#299EXOSOMES AND MICRO-RIBONUCLEIC ACIDS FOR TISSUE REGENERATION
#300ADVANCED CHIMERIC ANTIGEN RECEPTOR VECTORS FOR TARGETING SOLID TUMORS