110380 ⎘
Reverse transcribing RNA viruses; Details; Retroviridae; Lentivirus, not HIV, e.g. FIV, SIV; Use of virus, viral particle or viral elements as a vector virus or viral particle as vehicle, e.g. encapsulating small organic molecule
ENGINEERED ENVELOPED VECTORS AND METHODS OF USE THEREOF
#2SIRPalpha-SILENCED NATURAL KILLER (NK) CELLS
#3P21 Expressing Monocytes for Cancer Cell Therapy
#4MODIFIED RHABDOVIRUS GLYCOPROTEINS AND USES THEREOF
#5COMPOSITIONS AND METHODS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN HUMAN ANGELMAN SYNDROME
#6ENGINEERED PNMA PROTEINS AND DELIVERY SYSTEMS THEREOF
#7EBOLA PSEUDOTYPED VECTORS AND METHODS OF USE THEREOF
#8COMPOSITIONS AND METHODS FOR TREATING INTERLEUKIN 7 RECEPTOR DEFICIENCY
#9GENOMIC RNA PACKAGING ENHANCER ELEMENT
#10Methods of Treating Rheumatoid Arthritis Using RNA-Guided Genome Editing of HLA Gene
#11RETARGETED RETROVIRAL VECTORS AND COMPOSITIONS OR METHODS OF USE THEREOF
#12Methods and composition for gene delivery using an engineered viral particle
#13PERSONALIZED REDIRECTION AND REPROGRAMMING OF T CELLS FOR PRECISE TARGETING OF TUMORS
#14COMPOSITIONS AND METHODS FOR USING ALTERNATIVE SPLICING TO CONTROL SPECIFICITY OF GENE THERAPY
#15DAP10/12 BASED CARS ADAPTED FOR RUSH
#16ENGINEERED ENVELOPED VECTORS AND METHODS OF USE THEREOF
#17CRISPR-Cas13 crRNA Arrays
#18Novel Vectors and Uses Thereof
#19CHIMERIC ANTIGEN RECEPTOR TARGETING CLL1 AND USE THEREOF
#20CD25 PRE-SELECTIVE COMBINATION ANTI-HIV VECTORS, TARGETING VECTORS, AND METHODS OF USE
#21SIRPalpha-SILENCED NATURAL KILLER (NK) CELLS
#22VIRAL TARGETING OF HEMATOPOIETIC STEM CELLS
#23INDUCTION OF FUNCTIONAL ASTROCYTES FROM PLURIPOTENT STEM CELLS
#24PLURIPOTENT STEM CELL, NERVE CELL, AND APPLICATION THEREOF
#25CELLS EXPRESSING CHIMERIC ANTIGEN RECEPTORS AND CHIMERIC STIMULATING RECEPTORS AND USES THEREOF
#26Method for Transduction of T Cells in the Presence of Malignant Cells
#27Methods and composition for gene delivery using an engineered viral particle
#28METHOD FOR PREPARATION OF IMMORTALIZED STEM CELL LINE AND USE THEREOF
#29HEPATIC PRECURSOR-LIKE CELL LINE, CONSTRUCTION METHODS, AND APPLICATIONS IN THE FIELD OF THE BIOARTIFICIAL LIVERS
#30ENGINEERED IMMUNE CELLS COMPRISING A RECOGNITION MOLECULE
#31P21 Expressing Monocytes for Cancer Cell Therapy
#32Pharmaceutical Compositions Comprising Integration-Promoting Peptides
#33Lentivirus packaging system comprising a synthetic positive feedback loop
#34Compositions and methods to restore paternal UBE3A gene expression in human Angelman syndrome
#35Methods of improving vector transduction efficiency into T lymphocytes
#36Methods and composition for gene delivery using an engineered viral particle
#37MULTIPLEXED SHRNAS AND USES THEREOF
#38EXPRESSION VECTORS FOR CHIMERIC ENGULFMENT RECEPTORS, GENETICALLY MODIFIED HOST CELLS, AND USES THEREOF
#39Process for modifying human cell lines to produce factor VII
#40DAP10/12 BASED CARS ADAPTED FOR RUSH
#41VECTORS WITH PROMOTER AND ENHANCER COMBINATIONS FOR TREATING PHENYLKETONURIA
#42Methods to enhance myocardial regeneration and/or repair
#43Methods of treating rheumatoid arthritis using RNA-guided genome editing of HLA gene
#44CD25 PRE-SELECTIVE COMBINATION ANTI-HIV VECTORS, TARGETING VECTORS, AND METHODS OF USE
#45Compositions and methods for treating phenylketonuria
#46Genomic RNA packaging enhancer element
#47Lentivirus packaging system comprising a synthetic positive feedback loop
#48METHOD FOR PREPARING VIRAL PARTICLES WITH CYCLIC DINUCLEOTIDE AND USE OF SAID PARTICLES FOR TREATING CANCER
#49Lentiviral protein delivery system for RNA-guided genome editing
#50Multiplexed shRNAs and uses thereof
#51Methods of improving vector transduction efficiency into T lymphocytes
#52COMPOSITIONS AND METHODS FOR DIAGNOSING AND TREATING NUCLEOTIDE REPEAT DISORDERS
#53Pseudotyped lentiviral vectors
#54Genomic RNA packaging enhancer element
#55CD25 PRE-SELECTIVE COMBINATION ANTI-HIV VECTORS, TARGETING VECTORS, AND METHODS OF USE
#56WNT7A compositions and method of using the same
#57Methods for the treatment of nonalcoholic steatohepatitis