110523 ⎘
ssDNA viruses; Details; Parvoviridae; Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
SOD1 DUAL EXPRESSION VECTORS AND USES THEREOF
#2AAV-MEDIATED EXPRESSION USING A SYNTHETIC PROMOTER AND ENHANCER
#3Compositions for the Treatment of Infectious Disease Related Complications and Methods Thereof
#4VIRUS-DERIVED CONSTRUCT PLASMID LIBRARY AND CONSTRUCTION OF SAME
#5MODULATION OF NEURAL PATHWAYS
#6ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EXPRESSION IN INTERNEURONS
#7ENGINEERED VIRAL VECTORS WITH ENHANCED PACKAGING CAPACITY AND METHODS OF USING THE SAME
#8Products and Methods for Treatment of Amyotrophic Lateral Sclerosis
#9Products and Methods for Treatment of Amyotrophic Lateral Sclerosis
#10VIRAL VECTOR PRODUCTION SYSTEMS, ENGINEERED CELLS FOR VIRAL VECTOR PRODUCTION, AND METHODS OF USE THEREOF
#11Compositions and Methods for Altering Tissue Specificity and Improving AAV9-Mediated Gene Transfer
#12METHOD OF ALLELE SPECIFIC SILENCING FOR THE TREATMENT OF AUTOSOMAL DOMINANT CATECHOLAMINERGIC POLYMORPHIC VENTRICULAR TACHYCARDIA (CPVT)
#13AAV-MEDIATED EXPRESSION USING A SYNTHETIC PROMOTER AND ENHANCER
#14PROTOPARVOVIRUS AND TETRAPARVOVIRUS COMPOSITIONS AND METHODS FOR GENE THERAPY
#15SOD1 dual expression vectors and uses thereof
#16COMPOSITIONS USEFUL IN TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#17BIDIRECTIONAL DUAL PROMOTER EXPRESSION VECTORS AND USES THEREOF
#18COMPOSITIONS AND METHODS FOR THE TARGETING OF RHODOPSIN
#19COMPOSTIONS AND METHODS FOR NUCLEIC ACID TRANSFECTION USING CATIONIC POLYMERS AND STABILIZERS
#20ADENO-ASSOCIATED VIRUS VECTOR PLATFORM FOR DELIVERY OF KH902 (CONBERCEPT) AND USES THEREOF
#21Zinc Finger Protein Transcription Factors for Repressing Alpha-Synuclein Expression
#22GENE THERAPY FOR RETINAL DISEASE
#23OLIGONUCLEOTIDES AND METHODS FOR THE TREATMENT OF AGE-RELATED MACULAR DEGENERATION
#24GENE EDITING SYSTEM FOR CORRECTING SPLICING DEFECTS
#25ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EXPRESSION IN INTERNEURONS
#26De Novo Formation of the Biliary System by Hepatocyte Transdifferentiation
#27SynP159, a promoter for the expression of genes
#28Method of allele specific silencing for the treatment of autosomal dominant Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)
#29IMPROVED CLINICAL PARAMETERS BY EXPRESSION OF FACTOR VIII
#30Compositions and methods for altering tissue specificity and improving AAV9-mediated gene transfer
#31Modulation of neural pathways
#32Products and Methods for Treatment of Familial Amyotrophic Lateral Sclerosis
#33Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#34Gene therapies for lysosomal disorders
#35Gene therapies for lysosomal disorders
#36Gene therapies for lysosomal disorders
#37SOD1 dual expression vectors and uses thereof
#38Compositions and methods for altering tissue specificity and improving AAV9-mediated gene transfer
#39Products and methods for treatment of familial amyotrophic lateral sclerosis
#40AAV-mediated expression using a synthetic promoter and enhancer
#41Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#42SYNP159, a promoter for the specific expression of genes in rod photoreceptors
#43Baculovirus system for the expression of a gene therapy vector
#44Compositions and methods for altering tissue specificity and improving AAV9-mediated gene transfer
#45Multivalent PCV2 immunogenic compositions and methods of producing such compositions
#46Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#47Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#48Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#49RECOMBINANT VIRUS AND PREPARATIONS THEREOF
#50Multivalent PCV2 immunogenic compositions and methods of producing such compositions
#51Multivalent PCV2 immunogenic compositions and methods of producing such compositions
#52Baculovirus system for the expression of a gene therapy vector
#53Recombinant virus and preparations thereof
#54Compositions and methods for altering tissue specificity and improving AAV9-mediated gene transfer
#55Vaccines containing canine parvovirus genetic variants
#56Multivalent PCV2 immunogenic compositions and methods of producing such compositions
#57Method and Composition for Controlling Gene Expression
#58Crustaceans as production systems for therapeutic proteins
#59Vaccines containing canine parvovirus genetic variants
#60Multivalent PCV2 immunogenic compositions and methods of producing such compositions
#61Vaccines containing canine parvovirus genetic variants
#62MULTIVALENT PCV2 IMMUNOGENIC COMPOSITIONS AND METHODS OF PRODUCING SUCH COMPOSITIONS
#63Immunization regimen with E4-deleted adenovirus prime and E1-deleted adenovirus boost
#64Virus vectors and methods of making and administering the same
#65Virus vectors and methods of making and administering the same