110532 ⎘
ssDNA viruses; Details; Parvoviridae Demonstrated effect
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND THE TREATMENT OF MUSCULAR DYSTROPHY
#2ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR TARGETED GENE THERAPY
#3METHODS AND PHARMACEUTICAL COMPOSITION FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#4METHODS AND PHARMACEUTICAL COMPOSITIONS FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#5Adeno-associated virus compositions for targeted gene therapy
#6METHOD OF ALLELE SPECIFIC SILENCING FOR THE TREATMENT OF AUTOSOMAL DOMINANT CATECHOLAMINERGIC POLYMORPHIC VENTRICULAR TACHYCARDIA (CPVT)
#7COMPOSITIONS USEFUL IN TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#8BIDIRECTIONAL DUAL PROMOTER EXPRESSION VECTORS AND USES THEREOF
#9ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND THE TREATMENT OF MUSCULAR DYSTROPHY
#10Methods of vaccine administration
#11COMPOSITIONS AND METHODS FOR THE TARGETING OF RHODOPSIN
#12ADENO-ASSOCIATED VIRUS VECTOR PLATFORM FOR DELIVERY OF KH902 (CONBERCEPT) AND USES THEREOF
#13Zinc Finger Protein Transcription Factors for Repressing Alpha-Synuclein Expression
#14GENE THERAPY FOR RETINAL DISEASE
#15ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR TARGETED GENE THERAPY
#16METHODS AND PHARMACEUTICAL COMPOSITIONS FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#17GENE EDITING SYSTEM FOR CORRECTING SPLICING DEFECTS
#18METHODS AND PHARMACEUTICAL COMPOSITION FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#19Method of allele specific silencing for the treatment of autosomal dominant Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)
#20IMPROVED CLINICAL PARAMETERS BY EXPRESSION OF FACTOR VIII
#21Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#22Methods of vaccine administration
#23Adeno-associated virus compositions for targeted gene therapy
#24METHODS AND PHARMACEUTICAL COMPOSITIONS FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#25Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#26METHODS AND PHARMACEUTICAL COMPOSITION FOR THE TREATMENT AND THE PREVENTION OF CARDIOMYOPATHY DUE TO ENERGY FAILURE
#27Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#28Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#29Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#30Dry formulations of vaccines that are room temperature stable
#31Methods and pharmaceutical compositions for the treatment and the prevention of cardiomyopathy due to Friedreich ataxia
#32Methods of vaccine administration
#33Methods and pharmaceutical compositions for the treatment of cardiomyopathy due to friedreich ataxia
#34Vaccines containing canine parvovirus genetic variants
#35METHODS OF VACCINE ADMINISTRATION
#36Vaccines containing canine parvovirus genetic variants
#37Vaccines containing canine parvovirus genetic variants