110537 ⎘
ssDNA viruses; Details; Parvoviridae; Dependovirus, e.g. adenoassociated viruses Virus like particles [VLP]
ENGINEERED MUSCLE TARGETING COMPOSITIONS
#2LIVER-SPECIFIC VIRAL PROMOTERS AND METHODS OF USING THE SAME
#3NUCLEIC ACID CONSTRUCTS FOR VA RNA TRANSCRIPTION
#4METHODS FOR TREATING CANCER WITH HYPERACTIVE ADAR ENZYMES
#5ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#6ENGINEERED MUSCLE TARGETING COMPOSITIONS
#7FORMULATIONS FOR HIGHLY PURIFIED VIRAL PARTICLES
#8Method for separating full and empty AAV particles
#9Novel AAV rep ORFs and Rep polypeptides
#10COMPOSITIONS AND METHODS FOR THE MANAGEMENT AND TREATMENT OF PHENYLKETONURIA
#11VIRAL PARTICLES RETARGETED TO SKELETAL MUSCLE
#12GENE THERAPY
#13METHODS AND COMPOSITIONS FOR DELIVERY OF VIRAL VECTORS ACROSS THE BLOOD-BRAIN BARRIER
#14ANION EXCHANGE CHROMATOGRAPHY FOR RECOMBINANT AAV PRODUCTION
#15METHODS AND COMPOSITIONS FOR TARGETED GENE TRANSFER
#16HUMAN PAH EXPRESSION CASSETTE FOR TREATMENT OF PKU BY LIVER-DIRECTED GENE REPLACEMENT THERAPY
#17METHODS FOR DETECTING AAV
#18COMPOSITIONS AND METHODS FOR IMPEDING TRANSCRIPTION OF EXPANDED MICROSATELLITE REPEATS
#19TEMPLATED MUTAGENESIS AND NUCLEIC ACID SYNTHESIS
#20Methods for detecting AAV
#21ENGINEERED MUSCLE TARGETING COMPOSITIONS
#22METHODS FOR DETECTING AAV
#23SELF-INACTIVATING VECTORS FOR GENE EDITING
#24ANION-EXCHANGE CHROMATOGRAPHY METHODS FOR PURIFICATION OF RECOMBINANT ADENO-ASSOCIATED VIRUSES
#25TREATMENT OF COMPLEMENT-MEDIATED DISORDERS
#26METHOD FOR PRODUCING VIRUS PARTICLES
#27Methods and compositions for delivery of viral vectors across the blood-brain barrier
#28MICROTUBULE DESTABILIZER ADDITIVES TO INCREASE RECOMBINANT VIRAL VECTOR TITERS
#29METHOD FOR PURIFYING RECOMBINANT VIRAL PARTICLES
#30Methods for detecting AAV
#31AAV CAPSID DESIGNS
#32ENGINEERED AAV VECTORS
#33ADENO-ASSOCIATED VIRUS VECTORS
#34NOVEL RECOMBINANT ADENO-ASSOCIATED VIRUS CAPSIDS WITH ENHANCED HUMAN PANCREATIC TROPISM
#35Methods for using transcription-dependent directed evolution of AAV capsids
#36Methods for using transcription-dependent directed evolution of AAV capsids
#37Methods of predicting ancestral virus sequences and uses thereof
#38ENHANCED PURIFICATION OF ADENO-ASSOCIATED VIRUS TO MORE EFFECTIVELY REMOVE CONTAMINATING DNA
#39MATERIALS AND METHODS FOR VIRAL PURIFICATION
#40METHODS AND COMPOSITIONS FOR THE PURIFICATION OF ADENO-ASSOCIATED VIRUS
#41CLOSED-ENDED, LINEAR, DUPLEX ADENOASSOCIATED VIRUS DNA, AND USES THEREOF
#42CAPSID-MODIFIED RAAV VECTOR COMPOSITIONS AND METHODS THEREFOR
#43METHODS FOR USING TRANSCRIPTION-DEPENDENT DIRECTED EVOLUTION OF AAV CAPSIDS
#44CHARACTERIZATION OF GENE THERAPY VECTORS
#45NOVEL AAV3B VARIANTS THAT TARGET HUMAN HEPATOCYTES IN THE LIVER OF HUMANIZED MICE
#46Rescue of central and peripheral neurological phenotype of friedreich's ataxia by intravenous delivery
#47METHOD OF IN VIVO ADMINISTRATION OF THE CODING SEQUENCE OF THE SIRT6 GENE VIA ADENO-ASSOCIATED VIRUS
#48Online Native Mass Spectrometry Methods for Assaying Viral Particles
#49SYNTHETIC ADENO-ASSOCIATED VIRUS INVERTED TERMINAL REPEATS AND METHODS OF THEIR USE AS PROMOTERS
#50NOVEL AAV VARIANT
#51VIRAL CAPSID POLYPEPTIDES
#52FACTOR VIII POLYPEPTIDE
#53COMPOSITIONS AND METHODS OF INDUCING DIFFERENTIATION OF A HAIR CELL
#54ON-BIPOLAR CELL-SPECIFIC PROMOTERS FOR OCULAR GENE DELIVERY
#55METHOD FOR PURIFYING VIRUS OR VIRUS-LIKE PARTICLE
#56ENGINEERED MUSCLE TARGETING COMPOSITIONS
#57COMPOSITIONS AND METHODS FOR THE TREATMENT OF TAUOPATHY
#58ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#59CHARACTERIZATION OF GENE THERAPY VIRAL PARTICLES USING SIZE EXCLUSION CHROMATOGRAPHY AND MULTI-ANGLE LIGHT SCATTERING TECHNOLOGIES
#60MODIFIED ADENO-ASSOCIATED VIRUS (AAV) PARTICLES FOR GENE THERAPY
#61AAV VARIANTS WITH ENHANCED TROPISM
#62New Adeno-Associated Virus (AAV) Variants and Uses Thereof for Gene Therapy
#63ENHANCED TRANSDUCTION OF AAV VECTORS ENCODING MICRORNAS
#64Engineered muscle targeting compositions
#65COMPOSITIONS AND METHODS FOR PRODUCING ADENO-ASSOCIATED VIRAL VECTORS
#66AFFINITY-BASED MULTIPLEXING FOR LIVE-CELL MONITORING OF COMPLEX CELL POPULATIONS
#67INTRATHECAL AND INTRAVENOUS COMBINATION GENE THERAPY FOR THE TREATMENT OF INFANTILE BATTEN DISEASE
#68Nucleic acid constructs for VA RNA transcription
#69Human PAH expression cassette for treatment of PKU by liver-directed gene replacement therapy
#70Liver-specific viral promoters and methods of using the same
#71FORMULATIONS FOR HIGHLY PURIFIED VIRAL PARTICLES
#72PLASMID FREE AAV VECTOR PRODUCING CELL LINES
#73METHODS OF PREDICTING ANCESTRAL VIRUS SEQUENCES AND USES THEREOF
#74CODON-OPTIMIZED ABCB11 TRANSGENE FOR THE TREATMENT OF PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS TYPE 2 (PFIC2)
#75COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
#76Anion exchange chromatography for recombinant AAV production
#77COMPOSITIONS AND METHODS FOR TREATING WILSON'S DISEASE
#78ENGINEERED AAV CAPSIDS WITH INCREASED TROPISM AND AAV VECTORS COMPRISING THE ENGINEERED CAPSIDS AND METHODS OF MAKING AND USING SAME
#79COMPOSITIONS AND METHODS FOR MANUFACTURING GENE THERAPY VECTORS
#80Modified adeno-associated virus 5 capsids and uses thereof
#81Methods for using transcription-dependent directed evolution of AAV capsids
#82METHOD OF QUANTITATIVE MEASUREMENT OF PARTICLE CONTENT USING HYDRATED STATE IMAGING
#83Compositions and methods for impeding transcription of expanded microsatellite repeats
#84MODIFIED ADENO-ASSOCIATED VIRAL CAPSID PROTEINS FOR OCULAR GENE THERAPY AND METHODS OF USE THEREOF
#85MUTANT OF ADENO-ASSOCIATED VIRUS (AAV) CAPSID PROTEIN
#86ADENO-ASSOCIATED VIRAL VECTOR-MEDIATED GENE THERAPY FOR TREATING FRAGILE X-ASSOCIATED DISORDERS
#87GENE THERAPY VECTORS COMPRISING S/MAR SEQUENCES
#88RATIONALLY DESIGNED VIRUS-LIKE PARTICLES FOR MODULATION OF CHIMERIC ANTIGEN RECEPTOR (CAR)-T-CELL THERAPY
#89METHODS AND COMPOSITIONS FOR TREATMENT OF HEMOPHILIA
#90Methods for detecting AAV
#91AAV6 VARIANTS
#92Recombinant adeno-associated viruses encoding serpin peptides and uses thereof
#93Methods and compositions for delivery of viral vectors across the blood-brain barrier
#94Methods of predicting ancestral virus sequences and uses thereof
#95Closed-ended, linear, duplex adenoassociated virus DNA, and uses thereof
#96RESCUE OF CENTRAL AND PERIPHERAL NEUROLOGICAL PHENOTYPE OF FRIEDREICH'S ATAXIA BY INTRAVENOUS DELIVERY
#97Compositions and methods of treating Huntington's disease
#98TREATMENT OF COMPLEMENT-MEDIATED DISORDERS
#99Tropism-Modified Recombinant Viral Particles and Uses Thereof for the Targeted Introduction of Genetic Material into Human Cells
#100Methods of enhancing biological potency of baculovirus system-produced recombinant adeno-associated virus
#101Methods of predicting ancestral virus sequences and uses thereof
#102Assembly activating protein (AAP) and its use for the manufacture of parvovirus particles essentially consisting of VP3
#103Recombinant adeno-associated virus capsids with enhanced human pancreatic tropism
#104Mutant of adeno-associated virus (AAV) capsid protein
#105Method of quantitative measurement of particle content using hydrated state imaging
#106Materials and methods for treatment of Amyotrophic Lateral Sclerosis (ALS) and other related disorders
#107AAV capsid designs
#108REMOTE CONTROL OF LIGHT-TRIGGERED VIROTHERAPY
#109VIRAL NANOPARTICLES AND METHODS OF USE THEREOF
#110Methods of predicting ancestral virus sequences and uses thereof
#111MUTANT ADENO-ASSOCIATED VIRUS VIRIONS AND METHODS OF USE THEREOF
#112Methods of predicting ancestral virus sequences and uses thereof
#113Assembly activating protein (AAP) and its use for the manufacture of parvovirus particles essentially consisting of VP3
#114Methods of predicting ancestral virus sequences and uses thereof
#115METHODS AND COMPOSITIONS FOR GENE DELIVERY TO ON BIPOLAR CELLS
#116Anti-HER2 vaccine based upon AAV derived multimeric structures
#117Mutant adeno-associated virus virions and methods of use thereof
#118EXPRESSION OF VIRUS ENTRY INHIBITORS AND RECOMBINANT AAV THEREFOR
#119Virus vectors for highly efficient transgene delivery
#120Viral Vectors with Improved Properties
#121EXPRESSION OF VIRUS ENTRY INHIBITORS AND RECOMBINANT AAV THEREFOR
#122Assembly activating protein (AAP) and its use for the manufacture of parvovirus particles essentially consisting of VP3
#123PARVOVIRAL CAPSID WITH INCORPORATED GLY-ALA REPEAT REGION
#124Mutant adeno-associated virus virions and methods of use thereof
#125Expression of virus entry inhibitors and recombinant AAV therefor
#126Expression of virus entry inhibitors and recombinant AAV thereof
#127Viral vectors with improved properties