110546 ⎘
ssDNA viruses; Details; Parvoviridae; Dependovirus, e.g. adenoassociated viruses; Use of virus, viral particle or viral elements as a vector Special targeting system for viral vectors
RECOMBINANT AAVS WITH IMPROVED TROPISM AND SPECIFICITY
#2ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF
#3ENGINEERED MUSCLE TARGETING COMPOSITIONS
#4Gene Therapy for Genetic and Acquired Vasculopathies
#5ADENO-ASSOCIATED VIRUS (AAV) DIRECTED ANTIOXIDATIVE GENE THERAPY FOR THE PREVENTION, AMELIORATION, AND/OR TREATMENT OF HEARING LOSS
#6CAPSID VARIANTS AND METHODS OF USING THE SAME
#7RECOMBINANT AAV VECTORS FOR TREATING PROTEINOPATHIES IN CENTRAL NERVOUS SYSTEM
#8PRODUCTS AND METHODS FOR USE IN TREATING NDP-RELATED DISEASES
#9CAPSID POLYPEPTIDES AND METHODS OF USE THEREOF
#10OPTIMIZED CLN1 GENES AND EXPRESSION CASSETTES AND THEIR USE
#11ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#12ENGINEERED MUSCLE TARGETING COMPOSITIONS
#13ABCA4 TRANS-SPLICING MOLECULES
#14REDIRECTION OF TROPISM OF AAV CAPSIDS
#15MODIFIED COMPLEX PLATFORM OF ADENO-ASSOCIATED VIRUS WITH IMPROVED RATE OF EXPRESSION OF LOADED GENES AND REDUCED GENOTOXICITY
#16ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#17MUSCLE-SPECIFIC REGULATORY CASSETTES
#18CAPSID VARIANTS AND METHODS OF USING THE SAME
#19GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#20Virus-Ribonucleoprotein Conjugates
#21CAPSID VARIANTS AND METHODS OF USING THE SAME
#22ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT AND DECREASED LIVER ENRICHMENT
#23ADENO-ASSOCIATED VIRUS VIRION FOR TREATING ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#24MODIFIED CAPSID PROTEINS FOR ENHANCED DELIVERY OF PARVOVIRUS VECTORS
#25CHEMICALLY-MODIFIED ADENO-ASSOCIATED VIRUSES
#26RNAS TARGETING ACTIVIN A SUBUNITS
#27COMPOSITION FOR DELIVERING GENE TO BRAIN TISSUE AND USE THEREOF
#28MUTANT OF ADENO-ASSOCIATED VIRUS AND USE THEREOF
#29AAV VECTORS FOR RETINAL AND CNS GENE THERAPY
#30CAPSID VARIANTS AND METHODS OF USING THE SAME
#31RAAV VECTOR FOR THE TREATMENT OF COX20 DEFICIENCY
#32ADENO-ASSOCIATED VIRAL VECTORS FOR TARGETING BRAIN MICROVASCULATURE
#33METHOD FOR EXPRESSING A MUSCLE-SPECIFIC GENE AND CASSETTES FOR SAME
#34VIRAL PARTICLES RETARGETED TO SKELETAL MUSCLE
#35VECTORS AND METHODS FOR IN VIVO ANTIBODY PRODUCTION
#36ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#37SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS VECTOR AND ITS USE IN TREATMENT OF MUSCULAR DYSTROPHY
#38CAPSID VARIANTS AND METHODS OF USING THE SAME
#39MODIFIED VIRUSES AND VIRAL PARTICLES, METHODS OF MAKING, AND USES THEREOF
#40DUAL VECTOR SELF-INACTIVATING CRISPR/CAS9 SYSTEM
#41ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT AND/OR HEART ENRICHMENT
#42GENE SILENCING BY RECOMBINANT AAV-AMIRNA IN ALEXANDER DISEASE
#43ANTI-CD90 ANTIBODIES, BINDING FRAGMENTS, AND USES THEREOF
#44ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#45COMPOSITIONS AND METHODS FOR MUSCLE DISORDERS
#46CONTROLLED MUSCLE-SPECIFIC GENE DELIVERY
#47ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN THE CEREBELLUM AND A SECONDARY CELL TYPE
#48AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS WITH THE TRANSFERRIN RECEPTOR
#49ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RETINAL REGIONS
#50COMPOSITIONS AND METHODS FOR TREATING HER2 POSITIVE METASTATIC BREAST CANCER AND OTHER CANCERS
#51DOMINANT-NEGATIVE TUMOR NECROSIS FACTOR ALPHA ADENO-ASSOCIATED VIRUS GENE THERAPY
#52ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL GANGLION CELLS AND/OR RETINAL PIGMENT EPITHELIUM CELLS
#53FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION
#54Compositions Comprising Adeno-Associated Virus Chimera Capsid Proteins and Methods of Using the Same
#55CONJUGATION OF ADENO-ASSOCIATED VIRUSES
#56SELECTED AAV COMPOSITIONS HAVING PREFERRED BRAIN ENRICHMENT
#57GENE THERAPY FOR THE TREATMENT OF HT1
#58Treatments of Disorders of Myelin
#59CpG REDUCED FACTOR VIII VARIANTS, COMPOSITIONS AND METHODS AND USES FOR TREATMENT OF HEMOSTASIS DISORDERS
#60GENE THERAPEUTICS FOR TREATING BONE DISORDERS
#61THERAPEUTIC FACTORS FOR THE TREATMENT OF POLYQ DISEASES
#62GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTHMOGENIC CARDIOMYOPATHY
#63ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS AND METHODS OF USE THEREOF
#64COVALENTLY SURFACE MODIFIED ADENO-ASSOCIATED VIRUS PRODUCTION BY IN VITRO CONJUGATION, AND PURIFICATION OF COVALENTLY SURFACE MODIFIED ADENO-ASSOCIATED VIRUS
#65AAV CAPSID VARIANTS AND USES THEREOF
#66ADENO-ASSOCIATED VIRUS VECTOR VARIANTS FOR HIGH EFFICIENCY GENOME EDITING AND METHODS THEREOF
#67ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#68GENE THERAPY FOR THE TREATMENT OF WILSON'S DISEASE
#69METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS
#70AAV PARTICLES WITH MODIFIED INVERTED TERMINAL REPEATS FOR ENHANCED GENE EXPRESSION IN MUSCLE
#71VECTORS AND COMPOSITIONS FOR GENE AUGMENTATION OF CRUMBS COMPLEX HOMOLOGUE 1 (CRB1) MUTATIONS
#72MODIFIED AAV CAPSID PROTEIN AND USE THEREOF
#73MODIFIED ADENO-ASSOCIATED VIRUS VECTOR
#74AAV TRANSFER PLASMIDS
#75EXPRESSION CASSETTES FOR TREATING EPILEPSY AND NEUROPATHIC PAIN
#76ENGINEERED MUSCLE TARGETING COMPOSITIONS
#77ADENO-ASSOCIATED VIRUS VECTORS
#78ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#79TRANSGENE CASSETTES DESIGNED TO EXPRESS THE HUMAN CODON-OPTIMIZED GENE FMR1
#80ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#81COMPOSITIONS AND METHODS FOR DELIVERY OF AGENTS TO INNER EAR
#82CAPSID VARIANTS AND METHODS OF USING THE SAME
#83ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#84MODIFIED VIRAL PARTICLES FOR GENE THERAPY
#85ENGINEERED MUSCLE TARGETING COMPOSITIONS
#86ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#87FACTOR H VARIANTS FOR TREATMENT OF DISEASE
#88IN VIVO REPROGRAMMING OF PHOTORECEPTOR CELLS
#89ENGINEERED MUSCLE TARGETING COMPOSITIONS
#90GENE THERAPY FOR HEARING LOSS
#91ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF
#92KCNV2 Variants and Their Use
#93AAV CAPSID VARIANTS AND USES THEREOF
#94METHODS FOR EVALUATING TREATMENTS FOR BESTROPHINOPATHIES
#95VIRAL ADAPTORS AND USES THEREOF
#96ENGINEERED CENTRAL NERVOUS SYSTEM COMPOSITIONS
#97MODULATORS OF ADENO-ASSOCIATED VIRUS TRANSDUCTION AND USES THEREOF
#98ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED HEART AND SKELETAL MUSCLE ENRICHMENT
#99RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR TARGETED DELIVERY
#100CAPSID VARIANTS AND METHODS OF USING THE SAME
#101CAPSID VARIANTS AND METHODS OF USING THE SAME
#102CAPSID VARIANTS AND METHODS OF USING THE SAME
#103TREATMENT OF HEREDITARY ANGIOEDEMA WITH AAV GENE THERAPY VECTORS AND THERAPEUTIC FORMULATIONS
#104RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEPTIDES
#105AAV8 CAPSID VARIANTS WITH ENHANCED LIVER TARGETING
#106TARGETING MOIETIES PROMOTING TRANSDUCTION OF CENTRAL NERVOUS SYSTEM CELLS AND TISSUES AND METHODS OF USE
#107AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#108COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUROPATHY CAUSED BY ND4 MUTATION
#109Adeno-associated virus vectors modified to bind High-Density Lipoprotein
#110AAV Vectors Targeted to Oligodendrocytes
#111MODIFIED AAV CAPSIDS AND VECTORS
#112TREATMENT OF MUSCULAR DYSTROPHY
#113SLC13A5 GENE THERAPY VECTORS AND USES THEREOF
#114VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IGK SIGNAL SEQUENCE
#115ENGINEERING AAV VECTORS WITH IMPROVED CNS TARGETING
#116SYSTEMS AND METHODS FOR AN INTRANASAL DRUG DELIVERY SYSTEM
#117ENGINEERED TARGETING COMPOSITIONS FOR ENDOTHELIAL CELLS OF THE CENTRAL NERVOUS SYSTEM VASCULATURE AND METHODS OF USE THEREOF
#118AAV Vectors
#119NOVEL AAV SEROTYPES DERIVED FROM A LIBRARY SCREEN
#120COMPOSITIONS AND METHODS FOR ACHIEVING HIGH LEVELS OF TRANSDUCTION IN HUMAN LIVER CELLS
#121AAV VECTOR VARIANTS FOR OCULAR GENE DELIVERY
#122ADENO-ASSOCIATED VIRAL (AAV) VECTORS FOR TISSUE-TARGETED EXPRESSION OF THERAPEUTIC GENES
#123COMPOSITIONS AND METHODS FOR TREATING SENSORINEURAL HEARING LOSS USING STEREOCILIN DUAL VECTOR SYSTEMS
#124NOVEL COMPOSITIONS WITH BRAIN-SPECIFIC TARGETING MOTIFS AND COMPOSITIONS CONTAINING SAME
#125G-PROTEIN-GATED-K+ CHANNEL-MEDIATED ENHANCEMENTS IN LIGHT SENSITIVITY IN ROD-CONE DYSTROPHY (RCD)
#126COMPOSITIONS AND METHODS FOR TREATMENT OF CRX-MEDIATED RETINOPATHIES
#127CAPSID VARIANTS AND USES THEREOF
#128ADENO-ASSOCIATED VIRAL VECTORS FOR TRANSDUCTION OF COCHLEA
#129RECOMBINANT AAVS FOR DELIVERY TO CENTRAL NERVOUS SYSTEM AND BRAIN VASCULATURE
#130TISSUE-TARGETED MODIFIED AAV CAPSIDS AND METHODS OF USE THEREOF
#131GENE THERAPY
#132RATIONAL POLYPLOID AAV VIRIONS THAT CROSS THE BLOOD BRAIN BARRIER AND ELICIT REDUCED HUMORAL RESPONSE
#133VIRAL VECTORS WITH REDUCED IMMUNOGENICITY
#134ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND MICRORNA-29 AND THE TREATMENT OF MUSCULAR DYSTROPHY
#135AAVRH74 VECTORS FOR GENE THERAPY OF MUSCULAR DYSTROPHIES
#136VECTORIZED ANTI-CGRP AND ANTI-CGRPR ANTIBODIES AND ADMINISTRATION THEREOF
#137RECOMBINANT AAVS WITH IMPROVED TROPISM AND SPECIFICITY
#138COMPOSITIONS AND METHODS FOR USING ALTERNATIVE SPLICING TO CONTROL SPECIFICITY OF GENE THERAPY
#139Self-complementary AAV vectors carrying dominant negative RhoA and methods of use to treat ocular diseases
#140Brain Disease Therapy Enhancing Inhibition of GABAergic Neurons
#141ABCA4 TRANS-SPLICING MOLECULES
#142Compositions and methods of treating ocular diseases
#143Adeno-associated virus with engineered capsid
#144MUTATED ADENO-ASSOCIATED VIRAL CAPSID PROTEINS FOR CHEMICAL COUPLING OF LIGANDS, NANOPARTICLES OR DRUGS VIA THIOETHER BINDING AND PRODUCTION METHOD THEREOF
#145ENGINEERED MEGANUCLEASES THAT TARGET HUMAN MITOCHONDRIAL GENOMES
#146TELOMERASE REVERSE TRANSCRIPTASE-BASED THERAPIES
#147METHODS AND COMPOSITIONS FOR MODULATING THE INTERACTION BETWEEN ADENO-ASSOCIATED VIRUS (AAV) AND THE AAV RECEPTOR (AAVR) FOR ALTERED BIO-DISTRIBUTION OF AAV
#148LIGHT-CONTROLLED VIRAL TRANSDUCTION
#149GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTHMOGENIC CARDIOMYOPATHY
#150ABCA4 TRANS-SPLICING MOLECULES
#151ENGINEERED VIRAL CAPSIDS AND METHODS OF USE
#152NOVEL COMPOSITIONS WITH TISSUE-SPECIFIC TARGETING MOTIFS AND COMPOSITIONS CONTAINING SAME
#153Compositions and methods for treating non-age-associated hearing impairment in a human subject
#154LIVER DE-TARGETED RECOMBINANT AAV CAPSID PROTEINS
#155VARIANT TXNIP COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF DEGENERATIVE OCULAR DISEASES
#156METHODS OF TREATING METACHROMATIC LEUKODYSTROPHY
#157RATIONAL POLYPLOID ADENO-ASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF DISEASE
#158VECTORIZED ANTI-TNF-ALPHA ANTIBODIES FOR OCULAR INDICATIONS
#159AAV CAPSID DESIGNS
#160Optimized CLN1 genes and expression cassettes and their use
#161Capsid variants and methods of using the same
#162Modified viral particles for gene therapy
#163CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF
#164TREATMENT OF RPE65-ASSOCIATED EYE DISEASES AND DISORDERS
#165NOVEL ENGINEERED CAPSID SEROTYPE OF RECOMBINANT ADENO-ASSOCIATED VIRAL VECTOR WITH ENHANCED TRANSDUCTION EFFICIENCY AND WIDESPREAD DISTRIBUTION IN THE BRAIN
#166ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#167AAV VECTOR DELIVERY SYSTEMS
#168Engineered meganucleases that target human mitochondrial genomes
#169INSULIN RECEPTOR-MEDIATED ENHANCEMENT OF GENE TRANSFER
#170NUCLEIC ACID CONSTRUCTS AND USES THEREOF FOR TREATING SPINAL MUSCULAR ATROPHY
#171NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#172Methods for using transcription-dependent directed evolution of AAV capsids
#173Methods for using transcription-dependent directed evolution of AAV capsids
#174Adeno-associated virus variant capsids and methods of use thereof
#175ACTIVE DELIVERY OF NUCLEIC ACIDS AND PEPTIDES, METHODS AND USES
#176AAV VECTORS TARGETED TO THE CENTRAL NERVOUS SYSTEM
#177GENE EDITING TO IMPROVE JOINT FUNCTION
#178MINI-PROMOTER
#179Method for Engineering Novel Hybrid AAV Capsids Through Hyper Variable Regions Swapping
#180COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION OF GENE THERAPY VECTORS AND FOR REMOVING OR REDUCING IMMUNOGLOBULINS
#181MUSCLE-SPECIFIC NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USE THEREOF
#182BIFUNCTIONAL BRIDGING COMPOSITIONS FOR VIRAL TRANSDUCTION
#183ADENO-ASSOCIATED VIRUS VECTOR AND USE THEREOF
#184COMPOSITIONS AND METHODS FOR TREATING OCULAR DISORDERS
#185Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#186METHODS FOR USING TRANSCRIPTION-DEPENDENT DIRECTED EVOLUTION OF AAV CAPSIDS
#187TREATMENT OF RETINITIS PIGMENTOSA USING IMPROVED ENGINEERED MEGANUCLEASES
#188TREATMENT OF GLYCOGEN STORAGE DISEASE III
#189AAV Vector for Disrupting Coagulation Factor-Related Gene on Liver Genome
#190DISEASE CORRECTION BY DELIVERY OF AAV8 VECTORS EXPRESSING CODON OPTIMIZED NAGLU
#191Methods and Compositions for Treatment of Age-Related Dysfunction
#192COMPOSITIONS AND USES THEREOF FOR TREATMENT OF ANGELMAN SYNDROME
#193G-PROTEIN-GATED-K+ CHANNEL-MEDIATED ENHANCEMENTS IN LIGHT SENSITIVITY IN ROD-CONE DYSTROPHY (RCD)
#194Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy
#195TREATING AUTOSOMAL DOMINANT BESTROPHINOPATHIES AND METHODS FOR EVALUATING SAME
#196AAV CAPSIDS VARIANTS AND USES THEREOF
#197CAPSID-MODIFIED RAAV VECTOR COMPOSITIONS AND METHODS THEREFOR
#198GENE THERAPY
#199REDIRECTION OF TROPISM OF AAV CAPSIDS
#200High-transduction-efficiency rAAV vectors, compositions, and methods of use
#201ENGINEERED CRISPR/CAS13 SYSTEM AND USES THEREOF
#202PROSTATE TARGETING ADENO-ASSOCIATED VIRUS SEROTYPE VECTORS
#203COMPOSITIONS AND METHODS FOR TREATING NEUROFIBROMATIC DISORDERS
#204COMPOSITIONS AND METHODS FOR ENHANCING VISUAL FUNCTION
#205NOVEL AAV3B VARIANTS THAT TARGET HUMAN HEPATOCYTES IN THE LIVER OF HUMANIZED MICE
#206CRISPR/Cas-related methods and compositions for treating Leber's congenital amaurosis 10 (LCA10)
#207AAV CAPSID-PROMOTER INTERACTIONS AND CELL SELECTIVE GENE EXPRESSION
#208METHODS AND COMPOSITIONS FOR MODULATING THE INTERACTION BETWEEN ADENO-ASSOCIATED VIRUS (AAV) AND THE AAV RECEPTOR (AAVR) FOR ALTERED BIO-DISTRIBUTION OF AAV
#209Method for delivering RNA to neurons to treat herpes infections
#210KCNV2 variants and their use
#211ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#212COMPOSITIONS AND METHODS FOR THE TREATMENT OF TAUOPATHY
#213Adeno-associated virus virions with variant capsid and methods of use thereof
#214Adeno-associated virus virions with variant capsid and methods of use thereof
#215ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#216VIRAL PARTICLES FOR USE IN TREATING SYNUCLEINOPATHIES SUCH AS PARKINSON'S DISEASES BY GENE THERAPY
#217AAV CAPSID VARIANTS FOR GENE THERAPY
#218AAV VARIANTS WITH ENHANCED TROPISM
#219Modified AAV Capsid Proteins for Treatment of Arthritic Disease
#220Modified AAV capsid proteins and uses thereof
#221ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND MICRORNA-29 AND THE TREATMENT OF MUSCULAR DYSTROPHY
#222Adeno-associated virus variant capsids and methods of use thereof
#223Adeno-Associated Virus Virions with Variant Capsid and Methods of Use Thereof
#224Engineered muscle targeting compositions
#225COMPOSITIONS AND METHODS FOR TREATMENT OF CYSTIC FIBROSIS
#226MODIFIED VIRAL PARTICLES AND USES THEREOF
#227ENGINEERED MUSCLE TARGETING COMPOSITIONS
#228NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
#229PRODUCTION OF LARGE-SIZED QUASIDYSTROPHINS USING OVERLAPPING AAV VECTORS
#230RECOMBINANT ADENO-ASSOCIATED VIRUSES AND USES THEREOF
#231VIRAL VECTORS FOR THE TREATMENT OF DIABETES
#232MUTATED ADENO-ASSOCIATED VIRUS CAPSID PROTEINS, AAV PARTICLE COMPRISING THE SAME AND LIVER DIRECTED AAV VECTOR GENE THERAPY
#233ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#234SYSTEMS FOR EVOLVED ADENO-ASSOCIATED VIRUSES (AAVS) FOR TARGETED DELIVERY
#235Selective recovery
#236Materials and methods for delivering nucleic acids to cochlear and vestibular cells
#237MACHINE LEARNING ACCELERATED PROTEIN ENGINEERING THROUGH FITNESS PREDICTION
#238Modified capsid proteins for enhanced delivery of parvovirus vectors
#239REDIRECTION OF TROPISM OF AAV CAPSIDS
#240Adeno-associated virus variant capsids and methods of use thereof
#241Virus vectors for targeting ophthalmic tissues
#242Heterologous targeting peptide grafted AAVs
#243Adeno-associated virus virions with variant capsid and methods of use thereof
#244TELOMERASE REVERSE TRANSCRIPTASE-BASED THERAPIES
#245CAPSID-MODIFIED, RAAV3 VECTOR COMPOSITIONS AND METHODS OF USE IN GENE THERAPY OF HUMAN LIVER CANCER
#246COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
#247Variant adeno-associated viruses and methods of using
#248VIRAL VECTORS EXHIBITING IMPROVED GENE DELIVERY PROPERTIES
#249DIRECTED EVOLUTION
#250Isolation of novel AAV's and uses thereof
#251AAV vectors for retinal and CNS gene therapy
#252Rational polyploid adeno-associated virus vectors for the treatment of disease
#253COMPOSITIONS FOR TARGETING CONDUCTING AIRWAY CELLS COMPRISING ADENO-ASSOCIATED VIRUS CONSTRUCTS
#254MODIFIED AAV CAPSIDS AND USES THEREOF
#255Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#256Modified AAV capsid proteins and uses thereof
#257Use of Microvesicles in the Treatment of Medical Conditions
#258CAPSID-MODIFIED RAAV VECTORS AND METHODS OF USE
#259Gene therapeutics for treating bone disorders
#260AAV's and uses thereof
#261ADENO-ASSOCIATED VIRUS LIBRARY
#262MODIFIED RAAV CAPSID PROTEIN FOR GENE THERAPY
#263Adeno-associated virus virion for gene transfer to nervous system cells
#264Optimized CLN1 genes and expression cassettes and their use
#265AAV vectors
#266Treatment of glycogen storage disease III
#267Adeno-associated virus variant capsids and methods of use thereof
#268ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#269Mutated adeno-associated viral capsid proteins for chemical coupling of ligands, nanoparticles or drugs via thioether binding and production method thereof
#270AAV vectors targeted to the central nervous system
#271Systemic delivery of polypeptides
#272PEPTIDES AND NANOPARTICLES FOR INTRACELLULAR DELIVERY OF VIRUS
#273Chimeric capsids
#274Tropism-Modified Recombinant Viral Particles and Uses Thereof for the Targeted Introduction of Genetic Material into Human Cells
#275ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSIDS AND METHODS OF USE THEREOF
#276Rational polyploid adeno-associated virus vectors for the treatment of disease
#277Selective recovery
#278Recombinant AAV variants and uses thereof
#279Methods and compositions for treating Leber congenital amaurosis
#280CRISPR/CAS-related methods and compositions for treating Leber's Congenital Amaurosis 10 (LCA10)
#281Modified AAV capsid proteins and uses thereof
#282NOVEL RECOMBINANT ADENO-ASSOCIATED VIRUS CAPSIDS WITH ENHANCED HUMAN SKELETAL MUSCLE TROPISM
#283Heterologous targeting peptide grafted AAVS
#284Modified capsid proteins for enhanced delivery of parvovirus vectors
#285AAV vectors targeted to the central nervous system
#286AAV vectors targeted to oligodendrocytes
#287AAV capsid designs
#288Variant adeno-associated viruses and methods of using
#289Selective recovery
#290High-transduction-efficiency rAAV vectors, compositions, and methods of use
#291Isolation of novel AAV's and uses thereof
#292CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF
#293CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF
#294Use of microvesicles in the treatment of medical conditions
#295Synthetic combinatorial AAV capsid library for targeted gene therapy
#296Treatment of diseases by liver expression of an enzyme which has a deoxyribonuclease (DNase) activity
#297Method for delivering RNA to neurons to treat herpes infections
#298Adeno-associated virus virions with variant capsid
#299Adeno-associated virus vector delivery of B-sarcoglycan and microrna-29 and the treatment of muscular dystrophy
#300CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF