110548 ⎘
ssDNA viruses; Details; Parvoviridae; Dependovirus, e.g. adenoassociated viruses; Methods of production or purification of viral material relating to complementing cells and packaging systems for producing virus or viral particles
METHOD FOR THE PRODUCTION OF RECOMBINANT AAV PARTICLE PREPARATIONS
#2AAV-IDUA VECTOR FOR TREATMENT OF MPS I
#3AAV PARTICLES COMPRISING LIVER-TROPIC CAPSID PROTEIN AND ACID ALPHA-GLUCOSIDASE AND USE TO TREAT POMPE DISEASE
#4COMPOSITIONS AND METHODS FOR ADENO-ASSOCIATED VIRAL PRODUCTION
#5Polynucleotides for use in AAV production
#6METHOD FOR RELEASING VIRAL VECTORS
#7NUCLEIC ACID CONSTRUCTS FOR VA RNA TRANSCRIPTION
#8CAPSID VARIANTS AND METHODS OF USING THE SAME
#9RECOMBINANT AAV VECTORS FOR TREATING MUSCULAR DYSTROPHY
#10NOVEL DUAL HELPER PLASMID
#11TREATMENT OF CARDIOMYOPATHY WITH AAV GENE THERAPY VECTORS
#12CONTROLLED EXPRESSION OF VIRAL PROTEINS
#13CAPSID POLYPEPTIDES AND METHODS OF USE THEREOF
#14COMPOSITIONS AND METHODS FOR SELECTIVE GENE REGULATION
#15PLASMID FOR VIRUS-DERIVED STRUCTURE
#16Viral vector packaging cells with tunable virus genes to optimize vector production and quality
#17HYBRID AAV CAPSID AND USES THEREOF
#18ENHANCED DELIVERY OF VIRAL PARTICLES TO THE STRIATUM AND CORTEX
#19ADENO-ASSOCIATED VIRUS CAPSID HAVING TISSUE TROPISM AND USE THEREOF
#20COMPOSITION FOR TREATING RETINAL OR MACULAR DISEASES
#21AAV VECTORS PRODUCED BY INSECT CELLS COMPRISING REP52 AND REP78 CODING SEQUENCES WITH DIFFERENTIAL CODON BIASES
#22VECTORIZED ANTI-COMPLEMENT ANTIBODIES AND COMPLEMENT AGENTS AND ADMINISTRATION THEREOF
#23A CHIMERIC HELPER NUCLEIC ACID MOLECULE COMPRISING HELPER ELEMENTS FROM THREE DISTINCT HELPER VIRUSES
#24PRODUCT PREPARATION BASED ON APPLICATION OF SGRNA FOR THE TREATMENT OF HUNTINGTON'S DISEASE
#25METHOD FOR PRODUCING HIGH YIELD AND HIGH QUALITY RECOMBINANT ADENO-ASSOCIATED VIRUS
#26Novel AAV rep ORFs and Rep polypeptides
#27RECOMBINANT AAV HAVING AAV CLADE D AND CLADE E CAPSIDS AND COMPOSITIONS CONTAINING SAME
#28System for High-Level rAAV Production
#29ADENO-ASSOCIATED VIRUS GENE THERAPY PRODUCTS AND METHODS
#30A BIOENGINEERED AAV9 VECTOR CARRYING OPTIMIZED TRANSGENE FOR DUCHENNE MUSCULAR DYSTROPHY GENE THERAPY AND METHOD THEREOF
#31PRECISION RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR AND USE THEREOF
#32GENETIC REGULATORY ELEMENTS AND USES THEREOF
#33METHODS FOR MANUFACTURING VIRUSES AND VIRAL PARTICLES
#34IMPROVED RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTION
#35AAV VECTORS FOR GENE EDITING
#36NOVEL AAV CAPSID-MODIFIED STRAIN AND USE THEREOF
#37CAPSID VARIANTS AND METHODS OF USING THE SAME
#38VIRAL VECTOR PRODUCTION
#39COMPOUNDS FOR IMPROVEMENT OF VIRAL PRODUCTION
#40Tightly-Regulated Inducible Expression System for Production of Biologics Using Stable Cell Lines
#41Methods of Evaluating Virus-Producing Cells
#42EFFECTIVELY PACKAGING HIGH-QUALITY RAAV VECTORS BY MINICIRCLE DUAL TRANSFECTION
#43METHODS AND COMPOSITIONS FOR THE PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (rAAV) VECTORS
#44Insect cell-produced high potency AAV vectors with CNS-tropism
#45A SYSTEM FOR AN OCULAR GENE THERAPY AND A PROCESS FOR PREPARING THEREOF
#46ADENO-ASSOCIATED VIRUS PACKAGING VECTORS AND METHODS OF USING THE SAME
#47SELECTED AAV COMPOSITIONS HAVING PREFERRED BRAIN ENRICHMENT
#48EXOGENOUS GENE CONTROLLABLE EXPRESSION VIRUS PACKAGING VECTOR AND PACKAGING METHOD
#49HYBRID AAV CAPSIDS
#50THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC ACID ENCODING FACTOR VIII
#51Producer Cell Having Low Levels of VA-RNA
#52Higher yields and improved recombinant adeno-associated virus vectors by altering intracellular trafficking in producer cells.
#53GENE THERAPY FOR GAUCHER DISEASE
#54SYSTEMS AND METHODS FOR VIRAL TRANSFECTION OF CELLS IN A BIOREACTOR
#55OPTIMIZATION OF HEK293 SUSPENSION PLATFORM FOR IMPROVED rAAV TITERS
#56ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#57INTEGRATIVE PLASMID
#58MODIFIED BATCH AAV PRODUCTION SYSTEMS AND METHODS
#59ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VESTIBULAR SCHWANNOMA ASSOCIATED SYMPTOMS
#60ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VESTIBULAR SCHWANNOMA ASSOCIATED SYMPTOMS
#61COMPOSITIONS AND METHODS FOR RECOMBINANT AAV PRODUCTION
#62COMPOSITION AND METHODS FOR ADENO-ASSOCIATED VIRUS PRODUCING STABLE HUMAN EMBRYONIC KIDNEY-293 CELL LINES
#63EFFICIENT SYSTEM FOR PRODUCING ADENO-ASSOCIATED VIRUS (AAV) VECTOR
#64METHODS OF RAAV PACKAGING
#65METHOD OF INTRODUCING NUCLEIC ACID INTO CELL AND APPLICATION THEREOF
#66METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#67RECOMBINANT AAV VECTORS AND USES THEREOF
#68METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#69IMPROVED CELL LINES AND METHODS FOR THE PRODUCTION OF ADENO-ASSOCIATED VECTORS
#70AGENT FOR ENHANCING PRODUCTION OF VIRAL VECTOR AND METHOD FOR PRODUCING VIRAL VECTOR
#71INTEGRATIVE PLASMID
#72ADENO-ASSOCIATED VIRUS VECTOR VARIANTS FOR HIGH EFFICIENCY GENOME EDITING AND METHODS THEREOF
#73Stable Cell Lines for Inducible Production of rAAV Virions
#74TREATMENT OF ACQUIRED FOCAL EPILEPSY
#75AAV CAPSIDS FOR IMPROVED HEART TRANSDUCTION AND DETARGETING OF LIVER
#76AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#77Stable Cell Lines for Inducible Production of rAAV Virions
#78MODIFIED VECTOR, CONSTRUCTION METHOD, AND APPLICATION OF MODIFIED AAV-8 SEROTYPE FOR GENE TARGETING AND EXPRESSION
#79DELIVERY AND USE OF THE CRISPR-CAS SYSTEMS, VECTORS AND COMPOSITIONS FOR HEPATIC TARGETING AND THERAPY
#80CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND METHODS OF USING SAME
#81EXPRESSION CASSETTES FOR TREATING EPILEPSY AND NEUROPATHIC PAIN
#82LARGE SCALE ADENO-ASSOCIATED VIRUS PRODUCTION SYSTEMS
#83ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#84ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSES TYPE IV A
#85BACULOVIRUS VECTOR AND USE THEREOF IN PREPARATION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (rAAV) IN INSECT CELL
#86RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV) GENOME AND SINGLE-POLARITY RAAV VECTOR PACKAGED THEREBY
#87IN VIVO REPROGRAMMING OF PHOTORECEPTOR CELLS
#88GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
#89METHODS AND SYSTEMS FOR TRANSFECTING HOST CELLS
#90ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF
#91CELL LINES WITH IMPROVED AAV PRODUCTION CAPACITY
#92ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV)
#93PRODUCTION OF RECOMBINANT AAV VECTORS FOR TREATING MUSCULAR DYSTROPHY
#94Inducible AAV REP genes
#95STABLE PRODUCTION SYSTEMS FOR AAV VECTOR PRODUCTION
#96VIRAL VECTOR PRODUCTION
#97MODULATORS OF ADENO-ASSOCIATED VIRUS TRANSDUCTION AND USES THEREOF
#98HEK293 CELL LINE ADAPTED TO SERUM-FREE SUSPENSION CULTURE AND USE THEREOF
#99PRODUCER CELL, MANUFACTURING METHOD OF PRODUCER CELL, AND MANUFACTURING METHOD OF ADENO-ASSOCIATED VIRUS
#100ENGINEERED MUSCLE AND CENTRAL NERVOUS SYSTEM COMPOSITIONS
#101Method of Harvesting Biologics
#102RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEPTIDES
#103NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#104ENGINEERED PRODUCER CELL LINES AND METHODS OF MAKING AND USING THE SAME
#105Genetically Engineered Eukaryotic Cells and Cell Lines and Uses Thereof
#106SUSPENSION SYSTEM FOR ADENO ASSOCIATED VIRUS PRODUCTION
#107SELF-INACTIVATING VECTORS FOR GENE EDITING
#108STABLE PRODUCTION SYSTEMS FOR ADENO-ASSOCIATED VIRUS PRODUCTION
#109MODIFIED REP-CAP PLASMIDS AND USES THEREOF
#110GENETICALLY MODIFIED HIGH PRODUCTIVITY INSECT CELL LINES AND METHODS FOR OBTAINING SAME
#111AGENT FOR INDUCING VIRAL VECTOR PRODUCTION
#112Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism
#113ADENO-ASSOCIATED VIRUS CAPSID PROTEINS
#114Viral vector packaging cells made from cell hybrids
#115NOVEL AAV SEROTYPES DERIVED FROM A LIBRARY SCREEN
#116COMPOSITIONS AND METHODS FOR FORMATION AND SECRETION OF EXTRACELLULAR VESICLES AND AAV PARTICLES
#117NUCLEIC ACID CONSTRUCT FOR AIDS GENE THERAPY
#118VIRUS RECOVERY METHOD
#119AAV Manufacturing Methods
#120PRODUCTION OF ADENO-ASSOCIATED VIRUS VECTOR IN INSECT CELLS
#121Method for the Production of AAV
#122MODIFIED AAV CAPSIDS AND USES THEREOF
#123COMPOSITIONS AND METHODS FOR ADENO-ASSOCIATED VIRAL PRODUCTION
#124EXPRESSION CASSETTE FOR EXPRESSING GENE COMPRISING OVERLAPPING OPEN READING FRAMES IN INSECT CELL AND APPLICATION THEREOF
#125Insect cell production of parvoviral vectors with modified capsid proteins
#126METHODS FOR PRODUCING SINGLE INSECT CELL CLONES
#127ARSB VECTORS FOR TREATMENT OF MPS VI-ASSOCIATED BLINDNESS AND OTHER OCULAR MANIFESTATIONS
#128METHOD OF PRODUCING A RECOMBINANT VIRUS PARTICLE
#129MUTATION-INDEPENDENT GENE KNOCK-IN THERAPY TARGETING 5' UTR
#130VIRAL VECTOR CONSTRUCTS INCORPORATING DNA FOR INHIBITING TOLL LIKE RECEPTORS AND METHODS OF USING THE SAME
#131COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS AND/OR VISION LOSS
#132Method of Increasing the Function of an AAV Vector
#133METHODS OF REGULATING ADENO-ASSOCIATED VIRUS PRODUCTION
#134MICROTUBULE DESTABILIZER ADDITIVES TO INCREASE RECOMBINANT VIRAL VECTOR TITERS
#135HEK293T CELL STRAIN HAVING HIGH DISPERSIBILITY AND SCREENING METHOD THEREFOR
#136METHODS FOR ANALYSIS OF VIRAL CAPSID PROTEIN COMPOSITION
#137Mammalian cells and methods for engineering the same
#138GENERATION OF NEXT GENERATION RECOMBINANT AAV GENE THERAPY VECTORS THAT ADOPT 3D CONFORMATION
#139MAMMALIAN CELLS AND METHODS FOR ENGINEERING THE SAME
#140Cell hybrids as virus packaging cells for high efficiency production of gene therapy vectors and viral vaccines
#141VIRAL VECTOR PRODUCTION
#142METHOD OF MAKING RECOMBINANT AAVS
#143SUSPENSION MODE SEED TRAIN DEVELOPMENT FOR ADHERENT CELLS
#144VIRAL VECTOR-PRODUCING CELLS HAVING IMPROVED ABILITY TO PRODUCE VECTOR, METHOD FOR PRODUCING SAME AND METHOD FOR SELECTING SAME
#145METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#146VECTORS WITH MODIFIED INITIATION CODON FOR THE TRANSLATION OF AAV-REP78 USEFUL FOR PRODUCTION OF AAV
#147VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#148ENGINEERED CYCLIC PEPTIDES FOR ENHANCING VIRAL PRODUCTION
#149INDUCIBLE PROMOTER FOR VIRAL VECTOR PRODUCTION
#150INDUCIBLE PROMOTER FOR VIRAL VECTOR PRODUCTION
#151LIVER DE-TARGETED RECOMBINANT AAV CAPSID PROTEINS
#152CELL HYBRIDS AS HOST CELLS FOR HIGH EFFICIENCY PRODUCTION OF GENE THERAPY VECTORS AND VIRAL VACCINES
#153VARIANT TXNIP COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF DEGENERATIVE OCULAR DISEASES
#154IMPROVED ADENO-ASSOCIATED VIRUS (AAV) VECTOR AND USES THEREFOR
#155ABCD1 FOR TREATMENT OF NEURODISORDERS
#156PROCESS FOR MAKING A RECOMBINANT AAV LIBRARY
#157Inducible AAV REP genes
#158METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#159NOVEL ENGINEERED CAPSID SEROTYPE OF RECOMBINANT ADENO-ASSOCIATED VIRAL VECTOR WITH ENHANCED TRANSDUCTION EFFICIENCY AND WIDESPREAD DISTRIBUTION IN THE BRAIN
#160COMPOSITIONS AND METHODS FOR THE TREATMENT OF OCULAR DISEASES
#161METHODS OF PACKAGING MULTIPLE ADENO-ASSOCIATED VIRUS VECTORS
#162CELL CULTURE MEDIUM FOR USE IN PRODUCING GENE THERAPY PRODUCTS IN BIOREACTORS
#163ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VESTIBULAR SCHWANNOMA ASSOCIATED SYMPTOMS
#164METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#165NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#166METHODS AND COMPOSITIONS FOR THE PRODUCTION OF ADENO-ASSOCIATED VIRUS
#167CELL LINES FOR RECOMBINANT AAV PRODUCTION AND AAV-IMPLEMENTED PROTEIN PRODUCTION
#168METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#169Phagemid Vector
#170Method for Engineering Novel Hybrid AAV Capsids Through Hyper Variable Regions Swapping
#171COMPOSITIONS AND METHODS FOR REDUCING REVERSE PACKAGING OF CAP AND REP SEQUENCES IN RECOMBINANT AAV
#172COMPOSITIONS FOR TREATING FRIEDREICH’S ATAXIA
#173Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#174Suspension system for adeno associated virus production
#175GENE THERAPY OF NIEMANN-PICK DISEASE TYPE C
#176AAV PRODUCTION STRATEGY USING A CELL LINE EXPRESSING AN INDUCIBLE REP GENE
#177DEPLETION OF EXT1 EXPRESSION AND/OR ACTIVITY IMPROVES CELLULAR PRODUCTION OF BIOLOGICAL ENTITIES
#178METHODS AND COMPOSITIONS FOR PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUSES
#179RECOMBINANT AAV VECTORS WITH ALTERED IMMUNOGENCITY AND METHODS OF MAKING THE SAME
#180BACTERIAL HOST STRAINS
#181METHODS FOR ENHANCING RECOMBINANT ADENO-ASSOCIATED VIRUS YIELD
#182PREPARATION METHOD AND SYSTEM FOR RECOMBINANT ADENO-ASSOCIATED VIRUS, AND RECOMBINANT BACMID
#183RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS IN PLANTS
#184Dual helper plasmid
#185COMPOSITIONS AND METHODS FOR ENHANCING VISUAL FUNCTION
#186SYSTEM AND METHOD FOR PROCESSING VIRUS PREPARATIONS TO REDUCE HETEROGENEITY
#187ADENO-ASSOCIATED VIRUS PACKAGING SYSTEMS
#188Adeno-associated virus capsid proteins
#189ENHANCED DELIVERY OF VIRAL PARTICLES TO THE STRIATUM AND CORTEX
#190METHODS AND AAV VECTORS FOR IN VIVO TRANSDUCTION
#191VACCINE AND METHOD FOR TREATING CANCER
#192CONTROLLED EXPRESSION OF VIRAL PROTEINS
#193HOST SYSTEMS COMPRISING INHIBITORS OF A GENE-EDITING PROTEIN FOR PRODUCTION OF VIRAL VECTORS
#194IMPROVED PRODUCTION OF RECOMBINANT AAV USING EMBRYONATED AVIAN EGGS
#195RECOMBINANT HERPESVIRALES VECTOR
#196Methods for analysis of viral capsid protein composition
#197POTENCY ASSAYS FOR VIRAL VECTOR PRODUCTION
#198ADENO-ASSOCIATED VIRUS (AAV) PRODUCTION
#199AAV VECTORS PRODUCED BY INSECT CELLS COMPRISING REP52 AND REP78 CODING SEQUENCES WITH DIFFERENTIAL CODON BIASES
#200Adeno-Associated Virus Virions with Variant Capsid and Methods of Use Thereof
#201COMPOSITIONS AND METHODS FOR PRODUCING ADENO-ASSOCIATED VIRAL VECTORS
#202METHOD FOR PRODUCING NUCLEIC ACID-ENCAPSULATED AAV HOLLOW PARTICLE
#203Peptide-Modified Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism and Increased Muscle Transduction
#204CELLS FOR ENHANCED PRODUCTION OF ADENO-ASSOCIATED VIRUS
#205NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#206Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#207NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#208METHODS FOR THE MANUFACTURE OF RECOMBINANT VIRAL VECTORS
#209METHODS AND COMPOSITIONS FOR IMPROVING THE ASSEMBLY OF ADENO-ASSOCIATED VIRUSES (AAVs)
#210Inducible AAV System Comprising Cumate Operator Sequences
#211Stable cell lines for inducible production of rAAV virions
#212METHODS AND SYSTEMS OF PCR-BASED RECOMBINANT ADENO-ASSOCIATED VIRUS MANUFACTURE
#213COMPOSITIONS AND METHODS FOR SELECTIVE GENE REGULATION
#214Nucleic acid constructs for VA RNA transcription
#215VECTORS COMPRISING A NUCLEIC ACID ENCODING LYSOSOMAL ENZYMES FUSED TO A LYSOSOMAL TEARGETING SEQUENCE
#216AAV-based conditional expression system
#217MODIFIED ADENO-ASSOCIATED VIRAL VECTORS FOR USE IN GENETIC ENGINEERING
#218Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#219Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#220PLASMID FREE AAV VECTOR PRODUCING CELL LINES
#221CODON-OPTIMIZED ABCB11 TRANSGENE FOR THE TREATMENT OF PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS TYPE 2 (PFIC2)
#222EXPRESSION VECTORS FOR LARGE-SCALE PRODUCTION OF rAAV IN THE BACULOVIRUS/Sf9 SYSTEM
#223High titer recombinant AAV vector production in adherent and suspension cells
#224ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR IDS GENE TRANSFER AND METHODS OF USE THEREOF
#225COMPOSITIONS AND METHODS FOR MANUFACTURING GENE THERAPY VECTORS
#226AAV CAPSID PROTEINS FOR NUCLEIC ACID TRANSFER
#227RECOMBINANT AAV PRODUCTION IN MAMMALIAN CELLS
#228Recombinant adenoviral vector expressing Zika antigen with improved productivity
#229GENE THERAPY FOR THE TREATMENT OF GALACTOSEMIA
#230Methods and compositions for modifying assembly-activating protein (AAP)-dependence of viruses
#231Use of tonicifying agents to enhance recombinant adeno-associated virus yield
#232FURTHER IMPROVED AAV VECTORS PRODUCED IN INSECT CELLS
#233Codon-optimized acid alpha-glucosidase expression cassettes and methods of using same
#234DIRECTED EVOLUTION
#235Adenoassociated virus vectors for the treatment of mucopolysaccharidoses type IV A
#236SCALABLE METHOD FOR RECOMBINANT AAV PRODUCTION
#237Vector for the production of AAV particles
#238Vectors with modified initiation codon for the translation of AAV-Rep78 useful for production of AAV
#239METHODS AND COMPOSITIONS FOR ENGINEERED ASSEMBLY ACTIVATING PROTEINS (EAAPS)
#240COMPOSITIONS AND METHODS FOR TREATING DISEASES
#241Parvovirus Vector Production
#242Methods of packaging multiple adeno-associated virus vectors
#243SHRNA EXPRESSION CASSETTE, POLYNUCLEOTIDE SEQUENCE CARRYING SAME, AND APPLICATION THEREOF
#244Hybrid recombinant adeno-associated virus serotype between AAV9 and AAVrh74 with reduced liver tropism
#245MULTICISTRONIC EXPRESSION CONSTRUCTS
#246Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#247Methods for Adeno-Associated Viral Vector Production
#248METHODS OF AAV VECTOR PRODUCTION BY MODULATING DEUBIQUITINATING ENZYME ACTIVITY
#249METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#250INSECT CELL MANUFACTURED PARTIAL SELF-COMPLEMENTARY AAV GENOMES
#251VIRAL AND NON-VIRAL NANOPLASMID VECTORS WITH IMPROVED PRODUCTION
#252Delivery and use of the CRISPR-CAS systems, vectors and compositions for hepatic targeting and therapy
#253Method of increasing the function of an AAV vector
#254Engineered producer cell lines and methods of making and using the same
#255Adeno-associated virus compositions for PAH gene transfer and methods of use thereof
#256Methods for analysis of viral capsid protein composition
#257Column-based fully scalable rAAV manufacturing process
#258Adeno-associated virus compositions for PAH gene transfer and methods of use thereof
#259Inducible AAV Rep genes
#260Suspension system for adeno associated virus production
#261ADENO-ASSOCIATED VIRAL VECTORS FOR TREATING MUCOLIPIDOSIS TYPE II
#262Life-cycle-defective adenovirus helper viruses, their production and use for producing rAAV
#263Cancer treatment
#264METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#265Viral vector production
#266Adeno-associated virus (AAV) with modified phospholipase domain
#267Tropism-Modified Recombinant Viral Particles and Uses Thereof for the Targeted Introduction of Genetic Material into Human Cells
#268Vectors with modified initiation codon for the translation of AAV-REP78 useful for production of AAV
#269Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#270Methods for analysis of viral capsid protein composition
#271Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#272Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#273Cell culture methods involving HDAC inhibitors or rep proteins
#274Liver targeting adeno-associated viral vectors
#275Mammalian cells for producing adeno-associated viruses
#276Mutated rep encoding sequences for use in AAV production
#277Methods and compositions for modifying assembly-activating protein (AAP)-dependence of viruses
#278Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#279USE OF GLUCOCORTICOID ANALOGS TO ENHANCE RECOMBINANT ADENO-ASSOCIATED VIRUS YIELD
#280Adeno-associated virus compositions for PAH gene transfer and methods of use thereof
#281Intrathecal delivery of nucleic acid sequences encoding ABCD1 for treatment of adrenomyeloneuropathy
#282Adeno-associated virus virions with variant capsid
#283Method of increasing the function of an AAV vector
#284AAV vectors produced by insect cells comprising REP52 and REP78 coding sequences with differential codon biases
#285Vectors with modified initiation codon for the translation of AAV-Rep78 useful for production of AAV
#286Adeno-associated virus polynucleotides, polypeptides and virions
#287CELL LINE FOR RECOMBINANT PROTEIN AND/OR VIRAL VECTOR PRODUCTION
#288Therapeutic for treatment of diseases including the central nervous system
#289Production of oversized adeno-associated vectors
#290AAV-based conditional expression system
#291Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#292Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#293RECOMBINANT AAV PRODUCTION IN MAMMALIAN CELLS
#294AAV production in insect cells, methods and compositions therefor
#295Methods and compositions for modulating AAV infection
#296Methods for adeno-associated viral vector production
#297Phagemid vector
#298Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#299Vectors with modified initiation codon for the translation of AAV-Rep78 useful for production of AAV
#300AAV capsid proteins for nucleic acid transfer