117269 ⎘
Hydrolases acting on carbon-nitrogen bonds, other than peptide bonds (3.5) in cyclic amidines (3.5.4) Cytidine deaminase (3.5.4.5)
Engineered CasPhi2 Nucleases
#2FUSION PROTEIN CONTAINING CAS PROTEIN AND BACTERIAL TOXIN AND USE THEREOF
#3RNA-Guided Endonuclease Fusion Polypeptides and Methods of Use Thereof
#4RNA TICKERTAPE FOR RECORDING TRANSCRIPTIONAL HISTORIES OF CELLS
#5GENE EDITING FOR CONTROLLED EXPRESSION OF EPISOMAL GENES
#6COMPOSITIONS AND METHODS FOR REDUCING RNA LEVELS
#7NUCLEOBASE EDITORS AND METHODS OF USE THEREOF
#8CYTIDINE DEAMINASE VARIANTS FOR BASE EDITING
#9MODIFIED IMMUNE CELLS AND USES THEREOF
#10SINGLE BASE SUBSTITUTION PROTEIN, AND COMPOSITION COMPRISING SAME
#11GENOME EDITING TECHNIQUE
#12ANTIBODY-TARGETED ENZYMATIC CHEMOPROTECTION
#13TALE BASE EDITORS FOR GENE AND CELL THERAPY
#14ENGINEERED CYTIDINE DEAMINASES
#15COMPOSITIONS AND METHODS FOR ARTIFICIAL PROTOSPACER ADJACENT MOTIF (PAM) GENERATION
#16Cas12a Endonuclease Variants and Methods of Use
#17GENOME EDITING SYSTEMS FOR MULTIPLEXING POINT MUTATION INTRODUCTION IN LIVING CELLS
#18NOVEL ZINC FINGER FUSION PROTEINS FOR NUCLEOBASE EDITING
#19BASE EDITING-MEDIATED READTHROUGH OF PREMATURE TERMINATION CODONS (BERT)
#20REPROGRAMMABLE ISRB NUCLEASES AND USES THEREOF
#21EVOLVED CYTOSINE DEAMINASES AND METHODS OF EDITING DNA USING SAME
#22ENZYME, COMPLEX, RECOMBINANT VECTOR, THERAPEUTIC AGENT FOR GENETIC DISORDER, AND POLYNUCLEOTIDE
#23ISOLATED CAS13 PROTEINS, GENE EDITING SYSTEM BASED THEREON, AND USE THEREOF
#24RNA BASE EDITING COMPOSITIONS, SYSTEMS, METHODS AND USES THEREOF
#25SYSTEM FOR INDUCING MUTATION BASED ON OPTIMIZED ACTIVATION-INDUCED CYTIDINE DEAMINASE
#26NUCLEOBASE EDITORS AND USES THEREOF
#27NUCLEOBASE EDITORS COMPRISING GEOCAS9 AND USES THEREOF
#28REPROGRAMMABLE TNPB POLYPEPTIDES WITH MAZE DOMAINS AND USES THEREOF
#29CAS VARIANTS FOR GENE EDITING
#30COMPOSITIONS AND METHODS FOR TREATING A CONGENITAL EYE DISEASE
#31SYSTEMS METHODS, AND COMPOSITIONS FOR TARGETED NUCLEIC ACID EDITING
#32CRISPR-AID USING CATALYTICALLY INACTIVE RNA-GUIDED ENDONUCLEASE
#33FUSION PROTEINS, COMPOSITIONS COMPRISING THE SAME, AND METHODS OF USE THEREOF
#34EVOLVED CAS9 PROTEINS FOR GENE EDITING
#35MITOCHONDRIAL BASE EDITORS AND METHODS FOR EDITING MITOCHONDRIAL DNA
#36MODIFIED REGULATORY T CELLS AND METHODS OF USING THE SAME
#37BASE EDITORS AND USES THEREOF
#38METHOD FOR EDITING BANANA GENES
#39NOVEL RNA BASE EDITING COMPOSITIONS, SYSTEMS, METHODS AND USES THEREOF
#40REGENERATION OF SURFACE ANTIGEN-NEGATIVE CELLS
#41BASE EDITORS, COMPOSITIONS, AND METHODS FOR MODIFYING THE MITOCHONDRIAL GENOME
#42FUSION POLYPEPTIDES FOR GENETIC EDITING AND METHODS OF USE THEREOF
#43COMPOSITIONS AND METHODS FOR MULTIPLEX BASE EDITING IN HEMATOPOIETIC CELLS
#44EVOLVED DOUBLE-STRANDED DNA DEAMINASE BASE EDITORS AND METHODS OF USE
#45COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEREDITARY ANGIOEDEMA (HAE)
#46COMPOSITIONS AND METHODS FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY (SMA)
#47CYTIDINE DEAMINASES AND METHODS OF GENOME EDITING USING THE SAME
#48HIGHLY SENSITIVE IN VITRO ASSAYS TO DEFINE SUBSTRATE PREFERENCES AND SITES OF NUCLEIC-ACID BINDING, MODIFYING, AND CLEAVING AGENTS
#49BASE EDITING ENZYMES
#50Polynucleotides, Compositions, and Methods for Genome Editing
#51Modified Guide RNAs for Gene Editing
#52SYSTEMS, METHODS, AND COMPOSITIONS FOR RNA-GUIDED RNA-TARGETING CRISPR EFFECTORS
#53IMPROVED CYTOSINE TO GUANINE BASE EDITORS
#54Compositions and Methods for Analyzing Modified Nucleotides
#55CLEAVAGE-INACTIVE CAS12F1, CLEAVAGE-INACTIVE CAS12F1-BASED FUSION PROTEIN, CRISPR GENE-EDITING SYSTEM COMPRISING SAME, AND PREPARATION METHOD AND USE THEREOF
#56SYNTHETIC EXOSOMES (SE) FOR CNS DELIVERY OF CRISPR FOR GENE EDITING IN BRAIN DISORDERS
#57URACIL STABILIZING PROTEINS AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#58CHLOROPLAST CYTOSINE BASE EDITORS AND MITOCHONDRIA CYTOSINE BASE EDITORS IN PLANTS
#59METHOD FOR EDITING PLANT GENOME
#60REDIRECTING RISC FOR RNA EDITING
#61EVOLUTION OF CYTIDINE DEAMINASES
#62M6A-COUPLED EFFECTOR PROTEIN EXPRESSION SYSTEM AND METHODS OF MAKING AND USING SAME
#63HIGHLY SENSITIVE IN VITRO ASSAYS TO DEFINE SUBSTRATE PREFERENCES AND SITES OF NUCLEIC-ACID BINDING, MODIFYING, AND CLEAVING AGENTS
#64HIGH-THROUGHPUT METHODS FOR ANALYZING AND AFFINITY-MATURING AN ANTIGEN-BINDING MOLECULE
#65GENE THERAPY FOR TREATING BETA-HEMOGLOBINOPATHIES
#66ALTERED CYTIDINE DEAMINASES AND METHODS OF USE
#67NOVEL CRISPR ENZYMES, METHODS, SYSTEMS AND USES THEREOF
#68CHLOROPLAST CYTOSINE BASE EDITORS AND MITOCHONDRIA CYTOSINE BASE EDITORS IN PLANTS
#69ADENOSINE DEAMINASE BASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE IN A TARGET SEQUENCE
#70BASE EDITING OF TRANSTHYRETIN GENE
#71COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN AMYLOIDOSIS
#72CRISPR-ASSOCIATED BASED-EDITING OF THE COMPLEMENTARY STRAND
#73ZINC FINGER FUSION PROTEINS FOR NUCLEOBASE EDITING
#74CYTOSINE TO GUANINE BASE EDITOR
#75Small type II-D Cas proteins and methods of use thereof
#76INHIBITION OF UNINTENDED MUTATIONS IN GENE EDITING
#77Compositions and methods for detection and measurement of RNA modifications through targeted RNA editing
#78Polynucleotides, Compositions, and Methods for Genome Editing Involving Deamination
#79RNA-GUIDED ENDONUCLEASE FUSION POLYPEPTIDES AND METHODS OF USE THEREOF
#80RNA-GUIDED ENDONUCLEASE FUSION POLYPEPTIDES AND METHODS OF USE THEREOF
#81SMALL TYPE II-D CAS PROTEINS AND METHODS OF USE THEREOF
#82MINIATURIZED CYTIDINE DEAMINASE-CONTAINING COMPLEX FOR MODIFYING DOUBLE-STRANDED DNA
#83BASE EDITING APPROACHES FOR THE TREATMENT OF BETAHEMOGLOBINOPATHIES
#84NOVEL CRISPR ENZYMES, METHODS, SYSTEMS AND USES THEREOF
#85METHODS AND COMPOSITIONS FOR EVOLVING BASE EDITORS USING PHAGE-ASSISTED CONTINUOUS EVOLUTION (PACE)
#86IMPROVED RNA EDITING METHOD
#87MAGE-A1 SPECIFIC T CELL RECEPTOR AND USES THEREOF
#88METHOD FOR BASE EDITING IN PLANTS
#89COMPOSITIONS AND METHODS FOR BASE SPECIFIC MITOCHONDRIAL GENE EDITING
#90TARGETED BASE EDITING OF THE USH2A GENE
#91STAT3-TARGETED BASE EDITOR THERAPEUTICS FOR THE TREATMENT OF MELANOMA AND OTHER CANCERS
#92NUCLEOBASE EDITORS AND METHODS OF USE THEREOF
#93ENGINEERED BIFIDOBACTERIUM STRAINS COMPRISING A TRANSGENE
#94Inhibition of unintended mutations in gene editing
#95SYSTEMS AND METHODS FOR EVALUATING CAS9-INDEPENDENT OFF-TARGET EDITING OF NUCLEIC ACIDS
#96COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B
#97Compositions and methods for identifying RNA binding polypeptide targets
#98BASE-EDITING SYSTEMS
#99C-to-G Transversion DNA Base Editors
#100METHODS AND COMPOSITIONS FOR DNA BASE EDITING
#101SMALL TYPE II CAS PROTEINS AND METHODS OF USE THEREOF
#102Nucleobase editors comprising GeoCas9 and uses thereof
#103CRISPR TYPE V-U1 SYSTEM FROM MYCOBACTERIUM MUCOGENICUM AND USES THEREOF
#104BASE EDITORS WITH DIVERSIFIED TARGETING SCOPE
#105COILED-COIL MEDIATED TETHERING OF CRISPR/CAS AND EXONUCLEASES FOR ENHANCED GENOME EDITING
#106DETECTING METHYLCYTOSINE AND ITS DERIVATIVES USING S-ADENOSYL-L-METHIONINE ANALOGS (xSAMS)
#107RECOMBINANT RABIES VIRUSES FOR GENE THERAPY
#108Highly Efficient DNA Base Editors Mediated By RNA-Aptamer Recruitment For Targeted Genome Modification And Uses Thereof
#109Combinatorial Adenine and Cytosine DNA Base Editors
#110PROGRAMMABLE DNA BASE EDITING BY NME2CAS9-DEAMINASE FUSION PROTEINS
#111COMPOSITIONS AND METHODS FOR TARGETING MULTINUCLEATED CELLS
#112SINGLE BASE SUBSTITUTION PROTEIN, AND COMPOSITION COMPRISING SAME
#113NUCLEOBASE EDITORS AND USES THEREOF
#114TYPE VII CRISPR PROTEINS AND SYSTEMS
#115ADENOSINE DEAMINASE BASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE IN A TARGET SEQUENCE
#116COMPOSITIONS AND METHODS FOR IMPROVED GENE EDITING
#117CPF1 COMPLEXES WITH REDUCED INDEL ACTIVITY
#118HIGH-PRECISION BASE EDITORS
#119NUCLEOBASE EDITORS HAVING REDUCED OFF-TARGET DEAMINATION AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE TARGET SEQUENCE
#120MODIFIED IMMUNE CELLS HAVING ENHANCED ANTI-NEOPLASIA ACTIVITY AND IMMUNOSUPPRESSION RESISTANCE
#121Compositions and Methods for Improving Base Editing
#122Cas variants for gene editing
#123NUCLEOBASE EDITORS HAVING REDUCED NON-TARGET DEAMINATION AND ASSAYS FOR CHARACTERIZING NUCLEOBASE EDITORS
#124System and Method of Induced Mutant Protein Based on Activation-induced Cytidine Deaminase
#125Systems, methods, and compositions for RNA-guided RNA-targeting CRISPR effectors
#126Inhibition of unintended mutations in gene editing
#127RNA-guided endonuclease fusion polypeptides and methods of use thereof
#128METHODS OF SUPPRESSING PATHOGENIC MUTATIONS USING PROGRAMMABLE BASE EDITOR SYSTEMS
#129OPTIMIZED BASE EDITORS ENABLE EFFICIENT EDITING IN CELLS, ORGANOIDS AND MICE
#130RNA TICKERTAPE FOR RECORDING TRANSCRIPTIONAL HISTORIES OF CELLS
#131DIRECTED MODIFICATION OF RNA
#132MULTI-EFFECTOR NUCLEOBASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEIC ACID TARGET SEQUENCE
#133Evolution of cytidine deaminases
#134ENGINEERING B LYMPHOCYTES BY UTILIZING ENDOGENOUS ACTIVATION-INDUCED CYTIDINE DEAMINASE
#135Cytosine to guanine base editor
#136Compositions and methods for analyzing modified nucleotides
#137Base editors and uses thereof
#138Highly sensitive in vitro assays to define substrate preferences and sites of nucleic-acid binding, modifying, and cleaving agents
#139SYSTEMS, METHODS, AND COMPOSITIONS FOR TARGETED NUCLEIC ACID EDITING
#140Highly sensitive in vitro assays to define substrate preferences and sites of nucleic acid cleaving agents
#141CAS12B SYSTEMS, METHODS, AND COMPOSITIONS FOR TARGETED RNA BASE EDITING
#142Systems, methods, and compositions for targeted nucleic acid editing
#143Systems methods, and compositions for targeted nucleic acid editing
#144Compositions and methods for detection and measurement of RNA modifications through targeted RNA editing
#145Fusion proteins for improved precision in base editing
#146Systems, methods, and compositions for targeted nucleic acid editing
#147Cpf1 complexes with reduced indel activity
#148GENOMIC SEQUENCE MODIFICATION METHOD FOR SPECIFICALLY CONVERTING NUCLEIC ACID BASES OF TARGETED DNA SEQUENCE, AND MOLECULAR COMPLEX FOR USE IN SAME
#149CRISPR/CAS-CYTIDINE DEAMINASE BASED COMPOSITIONS, SYSTEMS, AND METHODS FOR TARGETED NUCLEIC ACID EDITING
#150RNA-guided endonuclease fusion polypeptides and methods of use thereof
#151Genomic sequence modification method for specifically converting nucleic acid bases of targeted DNA sequence, and molecular complex for use in same
#152Systems, methods, and compositions for targeted nucleic acid editing
#153Methods and compositions for evolving base editors using phage-assisted continuous evolution (PACE)
#154DNA WRITERS, MOLECULAR RECORDERS AND USES THEREOF
#155Highly sensitive in vitro assays to define substrate preferences and sites of nucleic-acid binding, modifying, and cleaving agents
#156Compositions and methods for identifying RNA binding polypeptide targets
#157ONCOLYTIC VIRUSES AND THERAPEUTIC MOLECULES
#158A METHOD OF ENGINEERING PRODRUG-SPECIFIC HYPERSENSITIVE T-CELLS FOR IMMUNOTHERAPY BY GENE EXPRESSION
#159Cas variants for gene editing
#160TARGETED MUTAGENESIS
#161METHODS AND KITS FOR DYNAMIC TARGETED HYPERMUTATION
#162Method for base editing in plants
#163Evolved Cas9 proteins for gene editing
#164Method for converting genome sequence of gram-positive bacterium by specifically converting nucleic acid base of targeted DNA sequence, and molecular complex used in same
#165Compositions and methods for analyzing modified nucleotides
#166Method for converting monocot plant genome sequence in which nucleic acid base in targeted DNA sequence is specifically converted, and molecular complex used therein
#167METHOD FOR MODIFYING GENOME SEQUENCE THAT SPECIFICALLY CONVERTS NUCLEOBASE OF TARGETED DNA SEQUENCE, AND MOLECULAR COMPLEX USED IN SAID METHOD
#168Triple-mode system for antibody maturation, surface display and secretion
#169Nucleobase editors and uses thereof
#170METHOD OF IDENTIFYING GENOME-WIDE OFF-TARGET SITES OF BASE EDITORS BY DETECTING SINGLE STRAND BREAKS IN GENOMIC DNA
#171Compositions and methods for analyzing modified nucleotides
#172Site-specific DNA base editing using modified APOBEC enzymes
#173DEAMINATION OF ORGANOPHOSPHORUS-NUCLEOSIDES
#174COMPOSITION AND METHOD FOR DIVERSIFYING POLYPEPTIDE LIBRARIES
#175Nucleobase editors and uses thereof
#176Genomic sequence modification method for specifically converting nucleic acid bases of targeted DNA sequence, and molecular complex for use in same
#177Cas variants for gene editing
#178Methods and compositions for discrimination between cytosine and modifications thereof, and for methylome analysis
#179Methods for nucleic acid editing
#180Fusions of Cas9 domains and nucleic acid-editing domains
#181METHODS FOR CORRECTING CASPASE-9 POINT MUTATIONS
#182Mutants of activation-induced cytidine deaminase (AID) and methods of use
#183Fusion Peptides That Bind to and Modify Target Nucleic Acid Sequences
#184Methods and compositions related to the structure and function of APOBEC3G
#185Modified cytosine deaminases
#186Three-dimensional structure of the APOBEC 2 structure, uses thereof, and methods for treating chronic and infectious diseases
#187Recombinant vector and use in gene therapy
#188Novel purified polypeptides from bacteria
#189Cytidine deaminase activators, deoxycytidine deaminase activators, Vif antagonists, and methods of screening for molecules thereof
#190Engineered adenosine deaminases and base editors thereof