117444 ⎘
in ketonic substances (3.7.1) Fumarylacetoacetase (3.7.1.2)
VIRAL VECTOR COMPOSITIONS AND METHODS OF USE THEREOF
#2GENE THERAPY FOR THE TREATMENT OF HT1
#3VECTORS AND METHODS OF USE
#4VECTORS AND METHODS OF USE
#5Fumarylacetoacetate hydrolase (FAH)-deficient and immunodeficient rats and uses thereof
#6Fumarylacetoacetate hydrolase (Fah)-deficient and immunodeficient rats and uses thereof