118427 ⎘
Ligases forming carbon-nitrogen bonds (6.3); Other carbon-nitrogen ligases (6.3.4) Argininosuccinate synthase (6.3.4.5)
MODULATION OF PROTEIN DEGRADATION
#2GENE THERAPY FOR TREATING CITRULLENEMIA
#3ASS1 Gene Insertion For The Treatment Of Citrullinemia Type I
#4IMPROVED BIOTECHNOLOGICAL METHOD FOR PRODUCING GUANIDINO ACETIC ACID (GAA) BY INACTIVATION OF AN AMINO ACID EXPORTER
#5METHOD FOR THE FERMENTATIVE PRODUCTION OF GUANIDINOACETIC ACID
#6IMPROVED BIOTECHNOLOGICAL METHOD FOR PRODUCING GUANIDINO ACETIC ACID (GAA) BY USING NADH-DEPENDENT DEHYDROGENASES
#7ARGINASE AND ARGININOSUCCINATE SYNTHASE FOR CANCER THERAPY
#8COMPOSITION AND METHODS INCLUDING RECOMBINANT VIRUSES MODULATING ARGININE BIOSYNTHESIS
#9Process of Preparing mRNA-Loaded Lipid Nanoparticles
#10GENE THERAPY FOR TREATING CITRULLENEMIA
#11METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF ARGININOSUCCINATE SYNTHETASE (ASS1)
#12MODULATION OF PROTEIN DEGRADATION
#13MRNA THERAPY FOR ARGININOSUCCINATE SYNTHETASE DEFICIENCY
#14GENE THERAPY VECTORS COMPRISING S/MAR SEQUENCES
#15FUSION PROTEINS
#16Stable gene transfer to proliferating cells
#17Gene therapy for treating citrullenemia
#18Process of Preparing mRNA-Loaded Lipid Nanoparticles
#19Compositions and methods relating to argininosuccinate synthetase
#20Stable Gene Transfer to Proliferating Cells
#21MRNA therapy for argininosuccinate synthetase deficiency
#22Compositions and methods relating to argininosucccinate synthetase
#23Polynucleotides targeted against the extended 5′-UTR region of argininosuccinate synthase and uses thereof