Cambridge, Massachusetts
United States
26
2026-06-04
The entities that hold a legal rights for patent applications filed by inventor PACKER Michael:
Michael PACKER from Cambridge, US has applied for patents for these inventions. The list has both pending applications and granted patents:
METHODS AND COMPOSITIONS FOR TREATING ALPHA-1 ANTITRYPSIN DEFICIENCY
#2 | 2026-04-23COMPOSITIONS AND METHODS FOR TREATING HEMOGLOBINOPATHIES
#3 | 2026-03-05COMPOSITIONS AND METHODS FOR TREATING HEMOGLOBINOPATHIES
#4 | 2025-04-03METHODS OF SUBSTITUTING PATHOGENIC AMINO ACIDS USING PROGRAMMABLE BASE EDITOR SYSTEMS
#5 | 2024-09-12GUIDE RNAS FOR CRISPR/CAS EDITING SYSTEMS
#6 | 2024-07-11COMPOSITIONS AND METHODS FOR EFFICIENT GENOME EDITING
#7 | 2024-04-25ADENOSINE DEAMINASE BASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE IN A TARGET SEQUENCE
#8 | 2024-04-11COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN AMYLOIDOSIS
#9 | 2023-11-30COMPOSITIONS AND METHODS FOR TREATING GLYCOGEN STORAGE DISEASE TYPE 1A
#10 | 2023-05-25METHODS OF EDITING SINGLE NUCLEOTIDE POLYMORPHISM USING PROGRAMMABLE BASE EDITOR SYSTEMS
#11 | 2023-05-11METHODS OF EDITING A DISEASE-ASSOCIATED GENE USING ADENOSINE DEAMINASE BASE EDITORS, INCLUDING FOR THE TREATMENT OF GENETIC DISEASE
#12 | 2023-04-27Compositions and methods for treating hemoglobinopathies
#13 | 2023-03-30COMPOSITIONS AND METHODS FOR TREATING ALPHA-1 ANTITRYPSIN DEFICIENCY
#14 | 2023-03-16MODIFIED IMMUNE CELLS HAVING ADENOSINE DEAMINASE BASE EDITORS FOR MODIFYING A NUCLEOBASE IN A TARGET SEQUENCE
#15 | 2023-03-09NOVEL NUCLEOBASE EDITORS AND METHODS OF USING SAME
#16 | 2023-03-09COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B
#17 | 2022-12-22Methods of substituting pathogenic amino acids using programmable base editor systems
#18 | 2022-11-24Compositions and methods for treating hemoglobinopathies
#19 | 2022-07-28COMPOSITIONS AND METHODS FOR TREATING HEMOGLOBINOPATHIES
#20 | 2022-04-28COMPOSITIONS AND METHODS FOR TREATING GLYCOGEN STORAGE DISEASE TYPE 1A
#21 | 2022-03-31SPLICE ACCEPTOR SITE DISRUPTION OF A DISEASE-ASSOCIATED GENE USING ADENOSINE DEAMINASE BASE EDITORS, INCLUDING FOR THE TREATMENT OF GENETIC DISEASE
#22 | 2021-12-09METHODS OF EDITING SINGLE NUCLEOTIDE POLYMORPHISM USING PROGRAMMABLE BASE EDITOR SYSTEMS
#23 | 2021-12-02METHODS OF SUPPRESSING PATHOGENIC MUTATIONS USING PROGRAMMABLE BASE EDITOR SYSTEMS
#24 | 2021-08-26Compositions and methods for treating hemoglobinopathies
#25 | 2021-08-19Compositions and methods for treating hemoglobinopathies
#26 | 2021-05-06Adenosine deaminase base editors and methods of using same to modify a nucleobase in a target sequence
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