20537 ⎘
Medicinal preparations containing organic active ingredients; Carbohydrates; Sugars; Derivatives thereof; Compounds having three or more nucleosides or nucleotides Double-stranded nucleic acids or oligonucleotides
POLMERIC TRANSFECTION REAGENTS TO DELIVER NUCLEIC ACIDS FOR HOST CELL MODIFICATION
#302CANCER THERAPIES COMPRISING PEPTIDE LOADED CXCR3- AND CCR5-INDUCING DENDRITIC CELLS AND CHEMOKINE MODULATORY AGENTS
#303AGENT FOR USE IN THE TREATMENT OF GLIOMA
#304COMPOSITION FOR ALLEVIATING HAIR GRAYING, PROMOTING HAIR GROWTH AND/OR PREVENTING OR ALLEVIATING HAIR LOSS, COMPRISING DOUBLE-STRANDED MIRNA AS ACTIVE INGREDIENT
#305NANOVESICLES DERIVED FROM CELL MEMBRANE, AND USE THEREOF
#306NOVEL THERAPEUTIC AGENT FOR SEPTICEMIA, AND A METHOD FOR SCREENING FOR SAME
#307CATIONIC LIPIDS AND COMPOSITIONS THEREOF
#308METHOD FOR PREVENTING OR TREATING DENTIN-DENTAL PULP DISEASE OR PERIODONTAL DISEASE, CONTAINING LPAR2 INHIBITOR
#309LIPID NANOPARTICLE (LNP) DELIVERY SYSTEMS AND USES THEREOF
#310GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#311RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#312BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#313Biodegradable lipids for the delivery of active agents
#314Uses of a saponin and method for its isolation
#315SEQUENTIAL INNATE AND ADAPTIVE IMMUNE MODULATION FOR CANCER TREATMENT
#316THERAPEUTIC TREATMENT OF TUMORS BY BLOCKING THE HEME SYNTHESIS-EXPORT AXIS
#317LIPID BILAYER COATED MESOPOROUS SILICA NANOPARTICLES WITH A HIGH LOADING CAPACITY FOR ONE OR MORE ANTICANCER AGENTS
#318HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#319Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors
#320RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#321LIPID-MODIFIED NUCLEIC ACID COMPOUNDS AND METHODS
#322IMMUNO-ONCOLOGY THERAPEUTIC COMPOSITION USING ADJUVANT INCLUDING LIPOPEPTIDES AND POLY (I:C)
#323COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#324BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#325METHODS AND COMPOSITIONS FOR TAU REDUCTION GENE THERAPY
#326BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#327COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#328COMPOSITIONS AND METHODS FOR PROMOTING THE MINERALIZATION OF BIOLOGICAL TISSUE
#329COMPOSITIONS AND METHODS TO TRANSFECT, TEST, AND TREAT SKIN CELLS
#330Methods Of Treating Metabolic Disorders And Cardiovascular Disease With Inhibin Subunit Beta E (INHBE) Inhibitors
#331SYNTHETIC DNA VECTORS AND METHODS OF USE
#332METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#333CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#334TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#335BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#336COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#337RAAV-BASED COMPOSITIONS AND METHODS
#338MULTITARGETING RNA COMPOSITIONS
#339NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF CNNM4 IN A CELL
#340SIRNA TARGETING 17Beta-HYDROXYSTEROID DEHYDROGENASE TYPE 13 AND SIRNA CONJUGATE
#341ANTIVIRAL NUCLEIC ACID
#342USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#343COMPOSITIONS FOR TREATING HEART DISEASE BY INHIBITING THE ACTION OF mAKAP-beta
#344STRONG POTENTIATION OF TLR3 AGONISTS EFFECTS USING FXR AGONISTS AS A COMBINED TREATMENT
#345Nucleic Acid Containing Nanoparticles
#346DETECTION AND TREATMENT OF AUTOIMMUNE DISORDERS
#347ANTI-CD96 ANTIBODIES AND METHODS OF USE THEREOF
#348Combination Therapies Comprising C/EBP Alpha saRNA
#349Treatment Of Type 2 Diabetes With Hepatocyte Nuclear Factor 4 Alpha (HNF4A) Agonists
#350COMBINATION THERAPIES TARGETING MITOCHONDRIAL BIOGENESIS FOR CANCER THERAPY
#351METHODS OF DETECTING AND REDUCING CANCER CELL CENTRAL NERVOUS SYSTEM COLONIZATION
#352ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#353COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#354METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES
#355MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#356Compositions and methods for detecting proteinopathies
#357METHODS AND COMPOSITIONS FOR DETECTION OF TUMOR DNA
#358DEOXYRIBONUCLEOSIDE OR DEOXYRIBONUCLEOTIDE HAVING NOVEL ARTIFICIAL BASE APPLICABLE TO SCREENING FOR DNA APTAMER, AND NUCLEIC ACID CONTAINING THE SAME
#359KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#360Non-liposomal systems for nucleic acid delivery
#361DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS
#362CATIONIC LIPID
#363STAUFEN1 AGENTS AND ASSOCIATED METHODS
#364PEGYLATED LIPID, LIPOSOME MODIFIED BY THE LIPID, PHARMACEUTICAL COMPOSITION CONTAINING THE LIPOSOME, FORMULATION AND APPLICATION THEREOF
#365THERAPY FOR METASTATIC UROTHELIAL CANCER WITH THE ANTIBODY-DRUG CONJUGATE, SACITUZUMAB GOVITECAN (IMMU-132)
#366EXTRACELLULAR VESICLES LOADED WITH AT LEAST TWO DIFFERENT NUCLEIC ACIDS
#367TMEM173 saRNA Compositions and Methods of Use
#368COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PCSK9
#369ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#370COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#371ADJUVANTED MUCOSAL SUBUNIT VACCINES FOR PREVENTING SARS-COV-2 TRANSMISSION AND INFECTION
#372LIPOSOME COMPOSITIONS AND METHODS OF USE THEREOF
#373Sequence specific antimicrobials
#374STING DEPENDENT ADJUVANTS
#375METHOD OF TREATING FATTY LIVER DISEASE
#376IN VITRO AND IN VIVO INTRACELLULAR DELIVERY OF SIRNA VIA SELF-ASSEMBLED NANOPIECES
#377CARBON NANOPARTICLE COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTICS TO SPECIFIC TARGET SITES
#378RNA SEQUENCE ADAPTATION
#379Lipid formulations for delivery of therapeutic agents
#380DOSAGES OF IMMUNOCONJUGATES OF ANTIBODIES AND SN-38 FOR IMPROVED EFFICACY AND DECREASED TOXICITY
#381OLIGONUCLEOTIDE FOR INDUCING N-EXON SKIPPING DURING REST MRNA PRECURSOR PROCESSING
#382Treatment Of Inflammation With Glucocorticoids And Angiopoietin-Like 7 (ANGPTL7) Inhibitors
#383COMPOSITIONS AND METHODS FOR MODIFYING A PREDETERMINED TARGET NUCLEIC ACID SEQUENCE
#384PEG LIPIDS AND LIPID NANOPARTICLES
#385ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE
#386ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT
#387HSD17B13 VARIANTS AND USES THEREOF
#388ANTI-CTLA4 ANTIBODIES AND METHODS OF MAKING AND USING THE SAME
#389DOSAGES OF IMMUNOCONJUGATES OF ANTIBODIES AND SN-38 FOR IMPROVED EFFICACY AND DECREASED TOXICITY
#390COMPOSITIONS AND METHODS FOR PREVENTION AND TREATMENT OF HEARING LOSS
#391DOSAGE REGIMEN FOR THE TREATMENT OF NASH
#392TREATMENT FOR AORTOPATHY
#393METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS
#394USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#395RNAI AGENT FOR INHIBITING HBV EXPRESSION AND USE THEREOF
#396RNAI CONJUGATES AND USES THEREOF
#397NUCLEIC ACIDS ENCODING HIV NEUTRALIZING ANTIBODIES AND USES THEREOF
#398COMPOSITION AND METHOD FOR REDUCING OXALATE LEVELS IN PATIENTS RECEIVING MAINTENANCE DIALYSIS
#399Compositions and methods for delivery of RNA
#400COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#401USE OF SODIUM TRANS-[TETRACHLORIDOBIS(1H-INDAZOLE)RUTHENATE(III)] FOR TREATING CANCERS
#402METHODS FOR PREPARATION OF PLASMID DNA/LIPID PARTICLES WITH DEFINED SIZE FOR IN VITRO AND IN VIVO TRANSFECTION
#403Advanced Cell-Permeable Peptide Carriers
#404METHODS FOR PROPHYLACTIC AND THERAPEUTIC TREATMENT OF 2019-nCoV USING siRNAs AGAINST ORF1AB and N-Protein
#405METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY
#406NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#407COMPOSITIONS AND METHODS FOR TREATING AGE-RELATED MACULAR DEGENERATION AND GEOGRAPHIC ATROPHY
#408METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS
#409METHODS AND COMPOSITIONS FOR REGENERATING HAIR CELLS IN THE INNER EAR OF ADULT MAMMALS
#410METHODS AND COMPOSITIONS FOR TREATING CANCERS USING ANTISENSE
#411TRPC3 AS A THERAPEUTIC TARGET FOR ALZHEIMER’S DISEASE
#412Novel Replicase Cycling Reaction (RCR) and the Related RdRP-Binding Site Designs Thereof
#413NANOPARTICLE COMPOSITIONS CONTAINING SUGAR FUNCTIONALIZED NUCLEIC ACID CARRIERS
#414COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#415COMPOSITIONS AND METHODS FOR IMPROVING IMMUNE SYSTEM FUNCTION
#416COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#417METHOD OF MODULATING CELL PROLIFERATION
#418MICELLAR NANOPARTICLES AND USES THEREOF
#419LOCALIZED THERAPY OF LOWER AIRWAYS INFLAMMATORY DISORDERS WITH PROINFLAMMATORY CYTOKINE INHIBITORS
#420TOXIC RNAi ACTIVE SEED SEQUENCES FOR KILLING CANCER CELLS
#421FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#422ENGINEERED ANTIBODIES AND USES THEREOF
#423HYALURONAN IS A DRIVER OF COVID-19 SEVERITY
#424ROR2 INHIBITORS AND USE THEREOF IN TREATING AND/OR PREVENTING CARTILAGE LOSS
#425ANTIBODIES BINDING TO GPRC5D
#426LIPID NANOPARTICLES FOR DELIVERING THERAPEUTICS TO LUNGS
#427Use of TLR agonist and anti-CD47 agent to enhance phagocytosis of cancer cells
#428THERAPEUTIC COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B
#429PHARMACEUTICAL COMPOSITION CONTAINING DOUBLE-STRANDED RIBONUCLEIC ACID INHIBITING EXPRESSION OF COMPLEMENT C5
#430MODULATION OF SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION 3 (STAT3) EXPRESSION
#431Lipids and compositions for the delivery of therapeutics
#432RNAi APPROACH FOR CROP PEST PROTECTION
#433ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#434Physiologically active substance carrier
#435COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING VIRAL INFECTIONS
#436Oligomers and oligomer conjugates
#437NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
#438OLIGONUCLEOTIDES FOR PMS2 MODULATION
#439TREATMENT OF HEMOPHILIA WITH FITUSIRAN
#440RECOMBINANT PROTEIN TARGETING PD-1 AND TGFBETA
#441TREATMENTS OF NON-ALCOHOLIC STEATOHEPATITIS (NASH)
#442AMINO ALCOHOL IONIZABLE LIPIDS
#443Exosome-targeted DNA vaccine
#444PEGYLATED LIPOSOMES FOR DELIVERY OF IMMUNOGEN-ENCODING RNA
#445METHODS AND COMPOSITIONS FOR WOUND HEALING
#446SYNERGISTIC INDUCTION OF IMMUNITY AGAINST RNA VIRUSES
#447Extrahepatic delivery
#448Albumin Production and Cell Proliferation
#449Compositions and methods for nanoparticle lyophile forms
#450SIRNA FOR TREATING HEPATIC FIBROSIS AND DELIVERY PREPARATION THEREOF
#451CHEMICAL MODIFICATIONS FOR INHIBITING EXPRESSION OF ALDH2
#452HUMAN ORAL MUCOSA STEM CELL SECRETOME
#453COMPOSITIONS AND METHODS FOR MODIFYING BACTERIAL GENE EXPRESSION
#454METHODS FOR TREATING ATHEROSCLEROTIC CARDIOVASCULAR DISEASE WITH LPA-TARGETED RNAi CONSTRUCTS
#455COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#456METHODS FOR PRODUCTION OF MSC-DERIVED EXOSOMES
#457SIRNA, MEDICAL COMPOSITIONS, AND METHODS FOR TREATING DIABETES USING THE SAME
#458NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#459SYNTHETIC LETHALITY AND THE TREATMENT OF CANCER
#460METHODS FOR X CHROMOSOME REACTIVATION
#461IMMUNOTHERAPY FOR THE TREATMENT OF CANCER
#462LIPID FORMULATIONS FOR NUCLEIC ACID DELIVERY
#463Modified short interfering nucleic acid (siNA) molecules and uses thereof
#464HOMOGENEOUS BETA-1,3-GLUCAN/NUCLEIC ACID COMPLEXES AND USE THEREOF
#465SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#466COMPOSITIONS AND METHODS OF USE OF CRISPR-CAS SYSTEMS IN NUCLEOTIDE REPEAT DISORDERS
#467METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#468METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#469Compositions and methods for delivery of RNA
#470EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
#471Methods for treating or preventing ophthalmological conditions
#472METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS
#473COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION
#474COMPOUNDS AND METHODS FOR REDUCING APOE EXPRESSION
#475Methods of altering bone growth by administration of Sost or Wise antagonist or agonist
#476Nucleic acid, composition and conjugate containing same, preparation method, and use thereof
#477COMPOSITIONS AND METHODS FOR TREATMENT OF SKIN CANCERS
#478RNAI THERAPY FOR HEPATITIS B VIRUS INFECTION
#479THERAPEUTIC AGENT FOR MALIGNANT MESOTHELIOMA AND METHOD FOR SELECTING PATIENT HAVING MALIGNANT MESOTHELIOMA
#480Nanostructured Gels Capable of Controlled Release of Encapsulated Agents
#481MRNA COMBINATION THERAPY FOR THE TREATMENT OF CANCER
#482RNA AND NUCLEIC ACID CARRIER INCLUDING THE SAME
#483USE OF PCSK9 INHIBITOR IN PREPARATION OF PRODUCT FOR TREATING MULTIPLE DISEASES
#484METHODS OF TREATMENT AND DIAGNOSIS OF MULTIPLE MYELOMA PROGRESSION
#485METHODS FOR INTRACELLULAR DELIVERY AND ENHANCED GENE TARGETING
#486SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#487METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY INHIBITION OF FBXO44
#488Delivery of hydrophobic active agent particles
#489RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES
#490TREATMENT OF CANCER USING A SMAD3 INHIBITOR
#491CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF
#492Amphiregulin gene-specific double-stranded oligonucleotide and composition for preventing and treating fibrosis-related diseases and respiratory diseases, comprising same
#493Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#494DISCONTINUOUS OLIGONUCLEOTIDE LIGANDS
#495Lipid nanoparticle compositions and methods for mRNA delivery
#496VESICLES COMPRISING A PTEN INHIBITOR AND USES OF SAME
#497HIGH-THROUGHPUT METHODS FOR PREPARING LIPID NANOPARTICLES AND USES THEREOF
#498Compositions of DNA Molecules, Methods of Making Therefor, and Methods of Use Thereof
#499Treatment of amyotrophic lateral sclerosis (ALS)
#500ANTIVIRAL SILENCING RNA MOLECULES, CHEMICALLY MODIFIED ANTIVIRAL SILENCING RNA MOLECULES WITH ENHANCED CELL PENETRATING ABILITIES, PHARMACEUTICAL COMPOSITIONS COMPRISING SAME AND USES THEREOF FOR TREATMENT OF VIRAL INFECTIONS
#501TARGETING OF LACTATE DEHYDROGENASE C, METHODS OF PREPARING SAME, AND METHODS OF USING SAME IN COMBINATION WITH ANTI-CANCER TREATMENTS
#502METHODS FOR ENCAPSULATING POLYNUCLEOTIDES INTO REDUCED SIZES OF LIPID NANOPARTICLES AND NOVEL FORMULATION THEREOF
#503METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#504Methods and Compositions for Diabetes Treatment and Beta-Cell Regeneration
#505METHODS OF TREATMENT AND DIAGNOSTIC OF PATHOLOGICAL CONDITIONS ASSOCIATED WITH INTENSE STRESS
#506Modified oligonucleotides
#507CFTR MRNA COMPOSITIONS AND RELATED METHODS AND USES
#508RNAS for complement inhibition
#509METHODS AND COMPOSITIONS FOR THE TREATMENT OF RETINOPATHY AND OTHER OCULAR DISEASES
#510LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#511USE OF APE1/REF-1 INHIBITORS FOR TREATMENT OF RETINAL DISEASES
#512COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3 EXPRESSION
#513METHODS FOR ENGINEERING NON-NEURONAL CELLS INTO NEURONS AND USING NEWLY ENGINEERED NEURONS TO TREAT NEURODEGENERATIVE DISEASES
#514MULTIMERIC OLIGONUCLEOTIDES WITH ENHANCED BIOACTIVITY
#515POLYPEPTIDES
#516Branched tail lipid compounds and compositions for intracellular delivery of therapeutic agents
#517Lipid nanoparticle compositions and methods for MRNA delivery
#518Lipid nanoparticle compositions and methods for MRNA delivery
#519Compositions and methods for treatment of sepsis-related disorders
#520METHODS FOR TREATING TRIPLE-NEGATIVE BREAST CANCER
#521FLT3 LIGAND FUSION PROTEINS AND METHODS OF USE
#522MOTOR NEURON-SPECIFIC EXPRESSION VECTORS
#523Methods of reducing severity of glaucoma by intravitreal administration of insulin-like growth factor binding protein-like 1 (IGFBPL1)
#524Methods of treatment using cholestosome vesicles for incorporation of molecules into chylomicrons
#525USE OF CIRCUTRN IN PREPARATION OF DRUG FOR TREATING HEART FAILURE, RECOMBINANT VECTOR, AND DRUG FOR TREATING HEART FAILURE
#526COMPOSITIONS FOR FLCN GENE MODULATION AND METHODS THEREOF
#527ENGINEERED MICROALGAE FEED TO IMPROVE HONEY BEE PATHOGEN RESISTANCE AND NUTRITION
#528AGENT FOR PREVENTING OR TREATING MUSCULAR DISEASE
#529NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF CNNM4 IN A CELL
#530COMPOSITIONS AND METHODS FOR TREATING AND PREVENTING INFLAMMATION
#531MODULATION OF FACTOR 11 EXPRESSION
#532Compositions and methods for inhibiting expression of transthyretin
#533BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#534MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT
#535METHODS AND COMPOSITIONS FOR TREATMENT OF APC-DEFICIENT CANCER
#536RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE
#537Use of PIWI-interacting RNA piR-hsa-211106
#538Lipid formulations for delivery of therapeutic agents
#539INTERFERON- INDUCING OLIGONUCLEOTIDE DUPLEXES AND METHODS OF USE
#540ALL-IN-ONE AAV VECTORS FOR TREATING CORONAVIRUS-INDUCED DISEASES
#541MODULATING IMMUNE RESPONSE
#542COMPOSITION FOR TREATING OR SENSITIZING INTERFERON BETA RESISTANT CANCER DISEASE COMPRISING CFLIP SIRNA
#543CONJUGATE OF DOUBLE-STRANDED SIRNA ANALOGUE
#544A DBAIT MOLECULE IN COMBINATION WITH KRAS INHIBITOR FOR THE TREATMENT OF CANCER
#545METHODS FOR INCREASING PLATELET COUNT BY INHIBITING BILIVERDIN IXBETA REDUCTASE
#546ANTIBODY-SN-38 IMMUNOCONJUGATES WITH A CL2A LINKER
#547USE OF STAT4 INHIBITORS FOR PREVENTION AND TREATMENT OF ALZHEIMER'S DISEASE
#548Compositions and Methods for Suppressing MSUT2
#549NANOPARTICLE PHARMACEUTICAL COMPOSITIONS WITH REDUCED NANOPARTICLE SIZE AND IMPROVED POLYDISPERSITY INDEX
#550RNA INTERFERENCE-INDUCING NUCLEIC ACID COMPRISING 8-OXOGUANINE, MODIFIED NUCLEIC ACID BINDING TO MICRORNA COMPRISING 8-OXOGUANINE, AND USES THEREOF
#551CIRCULAR RNA COMPOSITIONS AND METHODS
#552METHODS AND COMPOSITIONS FOR TREATING CORONAVIRUS INFECTIOUS DISEASE
#553Methods of altering bone growth by administration of Sost or Wise antagonist or agonist
#554LIPOSOMAL COMPOSITION FOR PREVENTING OR EARLY TREATMENT OF PATHOGENIC INFECTION
#555NUCLEIC ACID MOLECULE TARGETING MITF GENE AND USE THEREOF
#556SIRNA CONJUGATE, DOUBLE-STRANDED SIRNA CONJUGATE, SALT THEREOF AND APPLICATION THEREOF
#557POLYPEPTIDES DIRECTED AGAINST VIRAL INFECTION AND USES THEREOF
#558Pharmaceutical composition comprising organoid and anti-inflammatory agent for preventing or treating inflammatory bowel disease
#559GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS
#560AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#561DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR TREATING COVID-19 CONTAINING SAME
#562Compositions and methods of treating muscle atrophy and myotonic dystrophy
#563Compositions and methods of treating muscle atrophy and myotonic dystrophy
#564COMPOSITIONS AND METHODS FOR TREATING VIRUS INFECTION
#565COMPOSITIONS AND METHODS FOR PREVENTING AND/OR TREATING MICROBIAL INFECTIONS
#566RIG-I AGONISTS AND METHODS USING SAME
#567Nucleic acid molecules capable of modulating target gene expression and uses thereof
#568METHODS AND COMPOSITIONS FOR THE TREATMENT OF CANCER OR OTHER DISEASES
#569INHIBITION OF CYTOKINE-INDUCED SH2 PROTEIN IN NK CELLS
#570COMPOSITIONS AND METHODS FOR SILENCING DNAJC15 GENE EXPRESSION
#571Compositions and methods for dengue virus chimeric constructions in vaccines
#572ASPARAGINE SYNTHETASE INHIBITORS AND USES THEREOF
#573PHARMACEUTICAL COMBINATION AND USE THEREOF
#574COMBINATION THERAPIES TARGETING MITOCHONDRIAL BIOGENESIS FOR CANCER THERAPY
#575HETERONUCLEIC ACID CONTAINING MORPHOLINO NUCLEIC ACID
#576CHANNEL MODULATORS
#577Methods of treating metabolic disorders and cardiovascular disease with inhibin subunit beta E (INHBE) inhibitors
#578COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION
#579Anti-tissue factor antibodies, antibody-drug conjugates, and related methods
#580Nanotherapy Targeting RHAMM-Positive Tumors
#581Inhibitors of C5a for the Treatment of Corona Virus Infection
#582Oral Drug Delivery System and Method for Fabricating Thereof
#583COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#584EDIBLE PLANT-DERIVED MICROVESICLE COMPOSITIONS FOR DIAGNOSIS AND TREATMENT OF DISEASE
#585SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY
#586RNA FORMULATIONS FOR HIGH VOLUME DISTRIBUTION
#587Methods and compositions for genomic integration
#588TARGETING ALPHA3BETA1 INTEGRIN FOR TREATMENT OF CANCER AND OTHER DISEASES
#589SIRP-GAMMA TARGETED AGENTS FOR USE IN THE TREATMENT OF CANCER
#590COMPOSITIONS AND METHODS FOR TREATING OR AMELIORATING INFECTIONS
#591POLYMERIC NANOPARTICLES AND DERIVATIVES THEREOF FOR NUCLEIC ACID BINDING AND DELIVERY
#592CHIMERIC RECEPTOR BINDING PROTEINS RESISTANT TO PROTEOLYTIC DEGRADATION
#593Amino Acid Mediated Gene Delivery and Its Uses
#594LIPID MEMBRANE STRUCTURE FOR DELIVERY INTO SIRNA CELL
#595NOVEL USE OF ASPIRIN COMPOUND IN INCREASING NUCLEIC ACID EXPRESSION
#596METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1
#597LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#598RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#599Composition for preventing or treating keloids or hypertrophic scars
#600METHODS AND COMPOSITIONS FOR TREATMENT OF ATHEROSCLEROSIS