ClassID:

20537

A61K31/713 - page 2 - CPC Classification

Classification description:

Medicinal preparations containing organic active ingredients; Carbohydrates; Sugars; Derivatives thereof; Compounds having three or more nucleosides or nucleotides Double-stranded nucleic acids or oligonucleotides

Recent Application in this class:
#301
20240301138
2024-09-12

POLMERIC TRANSFECTION REAGENTS TO DELIVER NUCLEIC ACIDS FOR HOST CELL MODIFICATION

#302
20240299544
2024-09-12

CANCER THERAPIES COMPRISING PEPTIDE LOADED CXCR3- AND CCR5-INDUCING DENDRITIC CELLS AND CHEMOKINE MODULATORY AGENTS

#303
20240299538
2024-09-12

AGENT FOR USE IN THE TREATMENT OF GLIOMA

#304
20240299437
2024-09-12

COMPOSITION FOR ALLEVIATING HAIR GRAYING, PROMOTING HAIR GROWTH AND/OR PREVENTING OR ALLEVIATING HAIR LOSS, COMPRISING DOUBLE-STRANDED MIRNA AS ACTIVE INGREDIENT

#305
20240299302
2024-09-12

NANOVESICLES DERIVED FROM CELL MEMBRANE, AND USE THEREOF

#306
20240294910
2024-09-05

NOVEL THERAPEUTIC AGENT FOR SEPTICEMIA, AND A METHOD FOR SCREENING FOR SAME

#307
20240293574
2024-09-05

CATIONIC LIPIDS AND COMPOSITIONS THEREOF

#308
20240293440
2024-09-05

METHOD FOR PREVENTING OR TREATING DENTIN-DENTAL PULP DISEASE OR PERIODONTAL DISEASE, CONTAINING LPAR2 INHIBITOR

#309
20240293317
2024-09-05

LIPID NANOPARTICLE (LNP) DELIVERY SYSTEMS AND USES THEREOF

#310
20240287524
2024-08-29

GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#311
20240287515
2024-08-29

RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)

#312
20240285768
2024-08-29

BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS

#313
20240285767
2024-08-29

Biodegradable lipids for the delivery of active agents

#314
20240285708
2024-08-29

Uses of a saponin and method for its isolation

#315
20240285671
2024-08-29

SEQUENTIAL INNATE AND ADAPTIVE IMMUNE MODULATION FOR CANCER TREATMENT

#316
20240285670
2024-08-29

THERAPEUTIC TREATMENT OF TUMORS BY BLOCKING THE HEME SYNTHESIS-EXPORT AXIS

#317
20240285531
2024-08-29

LIPID BILAYER COATED MESOPOROUS SILICA NANOPARTICLES WITH A HIGH LOADING CAPACITY FOR ONE OR MORE ANTICANCER AGENTS

#318
20240279661
2024-08-22

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

#319
20240279660
2024-08-22

Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors

#320
20240279652
2024-08-22

RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES

#321
20240279267
2024-08-22

LIPID-MODIFIED NUCLEIC ACID COMPOUNDS AND METHODS

#322
20240277754
2024-08-22

IMMUNO-ONCOLOGY THERAPEUTIC COMPOSITION USING ADJUVANT INCLUDING LIPOPEPTIDES AND POLY (I:C)

#323
20240271136
2024-08-15

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#324
20240269289
2024-08-15

BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS

#325
20240269161
2024-08-15

METHODS AND COMPOSITIONS FOR TAU REDUCTION GENE THERAPY

#326
20240254491
2024-08-01

BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#327
20240254486
2024-08-01

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#328
20240252600
2024-08-01

COMPOSITIONS AND METHODS FOR PROMOTING THE MINERALIZATION OF BIOLOGICAL TISSUE

#329
20240252549
2024-08-01

COMPOSITIONS AND METHODS TO TRANSFECT, TEST, AND TREAT SKIN CELLS

#330
20240252528
2024-08-01

Methods Of Treating Metabolic Disorders And Cardiovascular Disease With Inhibin Subunit Beta E (INHBE) Inhibitors

#331
20240247284
2024-07-25

SYNTHETIC DNA VECTORS AND METHODS OF USE

#332
20240247266
2024-07-25

METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER

#333
20240247260
2024-07-25

CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE

#334
20240245784
2024-07-25

TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS

#335
20240245778
2024-07-25

BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS

#336
20240245618
2024-07-25

COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS

#337
20240240180
2024-07-18

RAAV-BASED COMPOSITIONS AND METHODS

#338
20240240177
2024-07-18

MULTITARGETING RNA COMPOSITIONS

#339
20240229041
2024-07-11

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF CNNM4 IN A CELL

#340
20240229037
2024-07-11

SIRNA TARGETING 17Beta-HYDROXYSTEROID DEHYDROGENASE TYPE 13 AND SIRNA CONJUGATE

#341
20240229035
2024-07-11

ANTIVIRAL NUCLEIC ACID

#342
20240226134
2024-07-11

USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS

#343
20240216466
2024-07-04

COMPOSITIONS FOR TREATING HEART DISEASE BY INHIBITING THE ACTION OF mAKAP-beta

#344
20240216364
2024-07-04

STRONG POTENTIATION OF TLR3 AGONISTS EFFECTS USING FXR AGONISTS AS A COMBINED TREATMENT

#345
20240216291
2024-07-04

Nucleic Acid Containing Nanoparticles

#346
20240210393
2024-06-27

DETECTION AND TREATMENT OF AUTOIMMUNE DISORDERS

#347
20240209082
2024-06-27

ANTI-CD96 ANTIBODIES AND METHODS OF USE THEREOF

#348
20240207304
2024-06-27

Combination Therapies Comprising C/EBP Alpha saRNA

#349
20240207204
2024-06-27

Treatment Of Type 2 Diabetes With Hepatocyte Nuclear Factor 4 Alpha (HNF4A) Agonists

#350
20240207202
2024-06-27

COMBINATION THERAPIES TARGETING MITOCHONDRIAL BIOGENESIS FOR CANCER THERAPY

#351
20240201194
2024-06-20

METHODS OF DETECTING AND REDUCING CANCER CELL CENTRAL NERVOUS SYSTEM COLONIZATION

#352
20240200075
2024-06-20

ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#353
20240190998
2024-06-13

COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS

#354
20240189612
2024-06-13

METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES

#355
20240189339
2024-06-13

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#356
20240183864
2024-06-06

Compositions and methods for detecting proteinopathies

#357
20240182948
2024-06-06

METHODS AND COMPOSITIONS FOR DETECTION OF TUMOR DNA

#358
20240182908
2024-06-06

DEOXYRIBONUCLEOSIDE OR DEOXYRIBONUCLEOTIDE HAVING NOVEL ARTIFICIAL BASE APPLICABLE TO SCREENING FOR DNA APTAMER, AND NUCLEIC ACID CONTAINING THE SAME

#359
20240182902
2024-06-06

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#360
20240182895
2024-06-06

Non-liposomal systems for nucleic acid delivery

#361
20240182892
2024-06-06

DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS

#362
20240180954
2024-06-06

CATIONIC LIPID

#363
20240180953
2024-06-06

STAUFEN1 AGENTS AND ASSOCIATED METHODS

#364
20240180951
2024-06-06

PEGYLATED LIPID, LIPOSOME MODIFIED BY THE LIPID, PHARMACEUTICAL COMPOSITION CONTAINING THE LIPOSOME, FORMULATION AND APPLICATION THEREOF

#365
20240180892
2024-06-06

THERAPY FOR METASTATIC UROTHELIAL CANCER WITH THE ANTIBODY-DRUG CONJUGATE, SACITUZUMAB GOVITECAN (IMMU-132)

#366
20240180847
2024-06-06

EXTRACELLULAR VESICLES LOADED WITH AT LEAST TWO DIFFERENT NUCLEIC ACIDS

#367
20240175033
2024-05-30

TMEM173 saRNA Compositions and Methods of Use

#368
20240175032
2024-05-30

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PCSK9

#369
20240175030
2024-05-30

ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#370
20240175017
2024-05-30

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#371
20240173399
2024-05-30

ADJUVANTED MUCOSAL SUBUNIT VACCINES FOR PREVENTING SARS-COV-2 TRANSMISSION AND INFECTION

#372
20240173258
2024-05-30

LIPOSOME COMPOSITIONS AND METHODS OF USE THEREOF

#373
20240165210
2024-05-23

Sequence specific antimicrobials

#374
20240158801
2024-05-16

STING DEPENDENT ADJUVANTS

#375
20240158791
2024-05-16

METHOD OF TREATING FATTY LIVER DISEASE

#376
20240156853
2024-05-16

IN VITRO AND IN VIVO INTRACELLULAR DELIVERY OF SIRNA VIA SELF-ASSEMBLED NANOPIECES

#377
20240156852
2024-05-16

CARBON NANOPARTICLE COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTICS TO SPECIFIC TARGET SITES

#378
20240150386
2024-05-09

RNA SEQUENCE ADAPTATION

#379
20240148875
2024-05-09

Lipid formulations for delivery of therapeutic agents

#380
20240148873
2024-05-09

DOSAGES OF IMMUNOCONJUGATES OF ANTIBODIES AND SN-38 FOR IMPROVED EFFICACY AND DECREASED TOXICITY

#381
20240148775
2024-05-09

OLIGONUCLEOTIDE FOR INDUCING N-EXON SKIPPING DURING REST MRNA PRECURSOR PROCESSING

#382
20240148774
2024-05-09

Treatment Of Inflammation With Glucocorticoids And Angiopoietin-Like 7 (ANGPTL7) Inhibitors

#383
20240148771
2024-05-09

COMPOSITIONS AND METHODS FOR MODIFYING A PREDETERMINED TARGET NUCLEIC ACID SEQUENCE

#384
20240148663
2024-05-09

PEG LIPIDS AND LIPID NANOPARTICLES

#385
20240141351
2024-05-02

ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE

#386
20240141348
2024-05-02

ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT

#387
20240141305
2024-05-02

HSD17B13 VARIANTS AND USES THEREOF

#388
20240141046
2024-05-02

ANTI-CTLA4 ANTIBODIES AND METHODS OF MAKING AND USING THE SAME

#389
20240139324
2024-05-02

DOSAGES OF IMMUNOCONJUGATES OF ANTIBODIES AND SN-38 FOR IMPROVED EFFICACY AND DECREASED TOXICITY

#390
20240139315
2024-05-02

COMPOSITIONS AND METHODS FOR PREVENTION AND TREATMENT OF HEARING LOSS

#391
20240139230
2024-05-02

DOSAGE REGIMEN FOR THE TREATMENT OF NASH

#392
20240139229
2024-05-02

TREATMENT FOR AORTOPATHY

#393
20240138418
2024-05-02

METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS

#394
20240131051
2024-04-25

USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS

#395
20240124879
2024-04-18

RNAI AGENT FOR INHIBITING HBV EXPRESSION AND USE THEREOF

#396
20240124875
2024-04-18

RNAI CONJUGATES AND USES THEREOF

#397
20240124561
2024-04-18

NUCLEIC ACIDS ENCODING HIV NEUTRALIZING ANTIBODIES AND USES THEREOF

#398
20240122960
2024-04-18

COMPOSITION AND METHOD FOR REDUCING OXALATE LEVELS IN PATIENTS RECEIVING MAINTENANCE DIALYSIS

#399
20240115728
2024-04-11

Compositions and methods for delivery of RNA

#400
20240115679
2024-04-11

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#401
20240115582
2024-04-11

USE OF SODIUM TRANS-[TETRACHLORIDOBIS(1H-INDAZOLE)RUTHENATE(III)] FOR TREATING CANCERS

#402
20240115513
2024-04-11

METHODS FOR PREPARATION OF PLASMID DNA/LIPID PARTICLES WITH DEFINED SIZE FOR IN VITRO AND IN VIVO TRANSFECTION

#403
20240110202
2024-04-04

Advanced Cell-Permeable Peptide Carriers

#404
20240110187
2024-04-04

METHODS FOR PROPHYLACTIC AND THERAPEUTIC TREATMENT OF 2019-nCoV USING siRNAs AGAINST ORF1AB and N-Protein

#405
20240102107
2024-03-28

METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY

#406
20240100166
2024-03-28

NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS

#407
20240100081
2024-03-28

COMPOSITIONS AND METHODS FOR TREATING AGE-RELATED MACULAR DEGENERATION AND GEOGRAPHIC ATROPHY

#408
20240100080
2024-03-28

METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS

#409
20240100079
2024-03-28

METHODS AND COMPOSITIONS FOR REGENERATING HAIR CELLS IN THE INNER EAR OF ADULT MAMMALS

#410
20240100078
2024-03-28

METHODS AND COMPOSITIONS FOR TREATING CANCERS USING ANTISENSE

#411
20240099277
2024-03-28

TRPC3 AS A THERAPEUTIC TARGET FOR ALZHEIMER’S DISEASE

#412
20240093286
2024-03-21

Novel Replicase Cycling Reaction (RCR) and the Related RdRP-Binding Site Designs Thereof

#413
20240093238
2024-03-21

NANOPARTICLE COMPOSITIONS CONTAINING SUGAR FUNCTIONALIZED NUCLEIC ACID CARRIERS

#414
20240093201
2024-03-21

COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS

#415
20240093200
2024-03-21

COMPOSITIONS AND METHODS FOR IMPROVING IMMUNE SYSTEM FUNCTION

#416
20240093199
2024-03-21

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE

#417
20240092915
2024-03-21

METHOD OF MODULATING CELL PROLIFERATION

#418
20240091151
2024-03-21

MICELLAR NANOPARTICLES AND USES THEREOF

#419
20240084306
2024-03-14

LOCALIZED THERAPY OF LOWER AIRWAYS INFLAMMATORY DISORDERS WITH PROINFLAMMATORY CYTOKINE INHIBITORS

#420
20240076677
2024-03-07

TOXIC RNAi ACTIVE SEED SEQUENCES FOR KILLING CANCER CELLS

#421
20240076664
2024-03-07

FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#422
20240076399
2024-03-07

ENGINEERED ANTIBODIES AND USES THEREOF

#423
20240075055
2024-03-07

HYALURONAN IS A DRIVER OF COVID-19 SEVERITY

#424
20240075053
2024-03-07

ROR2 INHIBITORS AND USE THEREOF IN TREATING AND/OR PREVENTING CARTILAGE LOSS

#425
20240067749
2024-02-29

ANTIBODIES BINDING TO GPRC5D

#426
20240065982
2024-02-29

LIPID NANOPARTICLES FOR DELIVERING THERAPEUTICS TO LUNGS

#427
20240058379
2024-02-22

Use of TLR agonist and anti-CD47 agent to enhance phagocytosis of cancer cells

#428
20240050463
2024-02-15

THERAPEUTIC COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B

#429
20240050462
2024-02-15

PHARMACEUTICAL COMPOSITION CONTAINING DOUBLE-STRANDED RIBONUCLEIC ACID INHIBITING EXPRESSION OF COMPLEMENT C5

#430
20240043837
2024-02-08

MODULATION OF SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION 3 (STAT3) EXPRESSION

#431
20240042039
2024-02-08

Lipids and compositions for the delivery of therapeutics

#432
20240041914
2024-02-08

RNAi APPROACH FOR CROP PEST PROTECTION

#433
20240041913
2024-02-08

ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF

#434
20240041771
2024-02-08

Physiologically active substance carrier

#435
20240035035
2024-02-01

COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING VIRAL INFECTIONS

#436
20240035032
2024-02-01

Oligomers and oligomer conjugates

#437
20240035030
2024-02-01

NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY

#438
20240035027
2024-02-01

OLIGONUCLEOTIDES FOR PMS2 MODULATION

#439
20240027478
2024-01-25

TREATMENT OF HEMOPHILIA WITH FITUSIRAN

#440
20240025967
2024-01-25

RECOMBINANT PROTEIN TARGETING PD-1 AND TGFBETA

#441
20240024349
2024-01-25

TREATMENTS OF NON-ALCOHOLIC STEATOHEPATITIS (NASH)

#442
20240024239
2024-01-25

AMINO ALCOHOL IONIZABLE LIPIDS

#443
20240018214
2024-01-18

Exosome-targeted DNA vaccine

#444
20240016736
2024-01-18

PEGYLATED LIPOSOMES FOR DELIVERY OF IMMUNOGEN-ENCODING RNA

#445
20240009342
2024-01-11

METHODS AND COMPOSITIONS FOR WOUND HEALING

#446
20240009276
2024-01-11

SYNERGISTIC INDUCTION OF IMMUNITY AGAINST RNA VIRUSES

#447
20240009225
2024-01-11

Extrahepatic delivery

#448
20240002854
2024-01-04

Albumin Production and Cell Proliferation

#449
20240000710
2024-01-04

Compositions and methods for nanoparticle lyophile forms

#450
20230416753
2023-12-28

SIRNA FOR TREATING HEPATIC FIBROSIS AND DELIVERY PREPARATION THEREOF

#451
20230416752
2023-12-28

CHEMICAL MODIFICATIONS FOR INHIBITING EXPRESSION OF ALDH2

#452
20230416745
2023-12-28

HUMAN ORAL MUCOSA STEM CELL SECRETOME

#453
20230405130
2023-12-21

COMPOSITIONS AND METHODS FOR MODIFYING BACTERIAL GENE EXPRESSION

#454
20230405040
2023-12-21

METHODS FOR TREATING ATHEROSCLEROTIC CARDIOVASCULAR DISEASE WITH LPA-TARGETED RNAi CONSTRUCTS

#455
20230390321
2023-12-07

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#456
20230390201
2023-12-07

METHODS FOR PRODUCTION OF MSC-DERIVED EXOSOMES

#457
20230383299
2023-11-30

SIRNA, MEDICAL COMPOSITIONS, AND METHODS FOR TREATING DIABETES USING THE SAME

#458
20230381319
2023-11-30

NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS

#459
20230374603
2023-11-23

SYNTHETIC LETHALITY AND THE TREATMENT OF CANCER

#460
20230372385
2023-11-23

METHODS FOR X CHROMOSOME REACTIVATION

#461
20230372384
2023-11-23

IMMUNOTHERAPY FOR THE TREATMENT OF CANCER

#462
20230372245
2023-11-23

LIPID FORMULATIONS FOR NUCLEIC ACID DELIVERY

#463
20230365970
2023-11-16

Modified short interfering nucleic acid (siNA) molecules and uses thereof

#464
20230365966
2023-11-16

HOMOGENEOUS BETA-1,3-GLUCAN/NUCLEIC ACID COMPLEXES AND USE THEREOF

#465
20230365965
2023-11-16

SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#466
20230365950
2023-11-16

COMPOSITIONS AND METHODS OF USE OF CRISPR-CAS SYSTEMS IN NUCLEOTIDE REPEAT DISORDERS

#467
20230364266
2023-11-16

METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION

#468
20230364265
2023-11-16

METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION

#469
20230364260
2023-11-16

Compositions and methods for delivery of RNA

#470
20230364127
2023-11-16

EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6

#471
20230364123
2023-11-16

Methods for treating or preventing ophthalmological conditions

#472
20230364122
2023-11-16

METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS

#473
20230357779
2023-11-09

COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION

#474
20230357770
2023-11-09

COMPOUNDS AND METHODS FOR REDUCING APOE EXPRESSION

#475
20230357377
2023-11-09

Methods of altering bone growth by administration of Sost or Wise antagonist or agonist

#476
20230355775
2023-11-09

Nucleic acid, composition and conjugate containing same, preparation method, and use thereof

#477
20230355656
2023-11-09

COMPOSITIONS AND METHODS FOR TREATMENT OF SKIN CANCERS

#478
20230355654
2023-11-09

RNAI THERAPY FOR HEPATITIS B VIRUS INFECTION

#479
20230355568
2023-11-09

THERAPEUTIC AGENT FOR MALIGNANT MESOTHELIOMA AND METHOD FOR SELECTING PATIENT HAVING MALIGNANT MESOTHELIOMA

#480
20230346946
2023-11-02

Nanostructured Gels Capable of Controlled Release of Encapsulated Agents

#481
20230346928
2023-11-02

MRNA COMBINATION THERAPY FOR THE TREATMENT OF CANCER

#482
20230346821
2023-11-02

RNA AND NUCLEIC ACID CARRIER INCLUDING THE SAME

#483
20230346773
2023-11-02

USE OF PCSK9 INHIBITOR IN PREPARATION OF PRODUCT FOR TREATING MULTIPLE DISEASES

#484
20230340604
2023-10-26

METHODS OF TREATMENT AND DIAGNOSIS OF MULTIPLE MYELOMA PROGRESSION

#485
20230340480
2023-10-26

METHODS FOR INTRACELLULAR DELIVERY AND ENHANCED GENE TARGETING

#486
20230340473
2023-10-26

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#487
20230340127
2023-10-26

METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY INHIBITION OF FBXO44

#488
20230338622
2023-10-26

Delivery of hydrophobic active agent particles

#489
20230338579
2023-10-26

RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES

#490
20230338361
2023-10-26

TREATMENT OF CANCER USING A SMAD3 INHIBITOR

#491
20230332179
2023-10-19

CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF

#492
20230332154
2023-10-19

Amphiregulin gene-specific double-stranded oligonucleotide and composition for preventing and treating fibrosis-related diseases and respiratory diseases, comprising same

#493
20230332153
2023-10-19

Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof

#494
20230332148
2023-10-19

DISCONTINUOUS OLIGONUCLEOTIDE LIGANDS

#495
20230330262
2023-10-19

Lipid nanoparticle compositions and methods for mRNA delivery

#496
20230330130
2023-10-19

VESICLES COMPRISING A PTEN INHIBITOR AND USES OF SAME

#497
20230330023
2023-10-19

HIGH-THROUGHPUT METHODS FOR PREPARING LIPID NANOPARTICLES AND USES THEREOF

#498
20230323418
2023-10-12

Compositions of DNA Molecules, Methods of Making Therefor, and Methods of Use Thereof

#499
20230323388
2023-10-12

Treatment of amyotrophic lateral sclerosis (ALS)

#500
20230323355
2023-10-12

ANTIVIRAL SILENCING RNA MOLECULES, CHEMICALLY MODIFIED ANTIVIRAL SILENCING RNA MOLECULES WITH ENHANCED CELL PENETRATING ABILITIES, PHARMACEUTICAL COMPOSITIONS COMPRISING SAME AND USES THEREOF FOR TREATMENT OF VIRAL INFECTIONS

#501
20230321135
2023-10-12

TARGETING OF LACTATE DEHYDROGENASE C, METHODS OF PREPARING SAME, AND METHODS OF USING SAME IN COMBINATION WITH ANTI-CANCER TREATMENTS

#502
20230320993
2023-10-12

METHODS FOR ENCAPSULATING POLYNUCLEOTIDES INTO REDUCED SIZES OF LIPID NANOPARTICLES AND NOVEL FORMULATION THEREOF

#503
20230313185
2023-10-05

METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY

#504
20230312728
2023-10-05

Methods and Compositions for Diabetes Treatment and Beta-Cell Regeneration

#505
20230305023
2023-09-28

METHODS OF TREATMENT AND DIAGNOSTIC OF PATHOLOGICAL CONDITIONS ASSOCIATED WITH INTENSE STRESS

#506
20230304008
2023-09-28

Modified oligonucleotides

#507
20230302039
2023-09-28

CFTR MRNA COMPOSITIONS AND RELATED METHODS AND USES

#508
20230302038
2023-09-28

RNAS for complement inhibition

#509
20230301967
2023-09-28

METHODS AND COMPOSITIONS FOR THE TREATMENT OF RETINOPATHY AND OTHER OCULAR DISEASES

#510
20230293723
2023-09-21

LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY

#511
20230293471
2023-09-21

USE OF APE1/REF-1 INHIBITORS FOR TREATMENT OF RETINAL DISEASES

#512
20230287425
2023-09-14

COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3 EXPRESSION

#513
20230287411
2023-09-14

METHODS FOR ENGINEERING NON-NEURONAL CELLS INTO NEURONS AND USING NEWLY ENGINEERED NEURONS TO TREAT NEURODEGENERATIVE DISEASES

#514
20230287406
2023-09-14

MULTIMERIC OLIGONUCLEOTIDES WITH ENHANCED BIOACTIVITY

#515
20230287098
2023-09-14

POLYPEPTIDES

#516
20230286903
2023-09-14

Branched tail lipid compounds and compositions for intracellular delivery of therapeutic agents

#517
20230285593
2023-09-14

Lipid nanoparticle compositions and methods for MRNA delivery

#518
20230285592
2023-09-14

Lipid nanoparticle compositions and methods for MRNA delivery

#519
20230285440
2023-09-14

Compositions and methods for treatment of sepsis-related disorders

#520
20230285439
2023-09-14

METHODS FOR TREATING TRIPLE-NEGATIVE BREAST CANCER

#521
20230279067
2023-09-07

FLT3 LIGAND FUSION PROTEINS AND METHODS OF USE

#522
20230277690
2023-09-07

MOTOR NEURON-SPECIFIC EXPRESSION VECTORS

#523
20230277623
2023-09-07

Methods of reducing severity of glaucoma by intravitreal administration of insulin-like growth factor binding protein-like 1 (IGFBPL1)

#524
20230277471
2023-09-07

Methods of treatment using cholestosome vesicles for incorporation of molecules into chylomicrons

#525
20230272417
2023-08-31

USE OF CIRCUTRN IN PREPARATION OF DRUG FOR TREATING HEART FAILURE, RECOMBINANT VECTOR, AND DRUG FOR TREATING HEART FAILURE

#526
20230272401
2023-08-31

COMPOSITIONS FOR FLCN GENE MODULATION AND METHODS THEREOF

#527
20230272395
2023-08-31

ENGINEERED MICROALGAE FEED TO IMPROVE HONEY BEE PATHOGEN RESISTANCE AND NUTRITION

#528
20230272386
2023-08-31

AGENT FOR PREVENTING OR TREATING MUSCULAR DISEASE

#529
20230265438
2023-08-24

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF CNNM4 IN A CELL

#530
20230265199
2023-08-24

COMPOSITIONS AND METHODS FOR TREATING AND PREVENTING INFLAMMATION

#531
20230263822
2023-08-24

MODULATION OF FACTOR 11 EXPRESSION

#532
20230257740
2023-08-17

Compositions and methods for inhibiting expression of transthyretin

#533
20230256098
2023-08-17

BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS

#534
20230256001
2023-08-17

MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT

#535
20230250433
2023-08-10

METHODS AND COMPOSITIONS FOR TREATMENT OF APC-DEFICIENT CANCER

#536
20230250431
2023-08-10

RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE

#537
20230250425
2023-08-10

Use of PIWI-interacting RNA piR-hsa-211106

#538
20230248831
2023-08-10

Lipid formulations for delivery of therapeutic agents

#539
20230242918
2023-08-03

INTERFERON- INDUCING OLIGONUCLEOTIDE DUPLEXES AND METHODS OF USE

#540
20230242914
2023-08-03

ALL-IN-ONE AAV VECTORS FOR TREATING CORONAVIRUS-INDUCED DISEASES

#541
20230242630
2023-08-03

MODULATING IMMUNE RESPONSE

#542
20230241176
2023-08-03

COMPOSITION FOR TREATING OR SENSITIZING INTERFERON BETA RESISTANT CANCER DISEASE COMPRISING CFLIP SIRNA

#543
20230235330
2023-07-27

CONJUGATE OF DOUBLE-STRANDED SIRNA ANALOGUE

#544
20230235327
2023-07-27

A DBAIT MOLECULE IN COMBINATION WITH KRAS INHIBITOR FOR THE TREATMENT OF CANCER

#545
20230233712
2023-07-27

METHODS FOR INCREASING PLATELET COUNT BY INHIBITING BILIVERDIN IXBETA REDUCTASE

#546
20230233694
2023-07-27

ANTIBODY-SN-38 IMMUNOCONJUGATES WITH A CL2A LINKER

#547
20230233595
2023-07-27

USE OF STAT4 INHIBITORS FOR PREVENTION AND TREATMENT OF ALZHEIMER'S DISEASE

#548
20230233594
2023-07-27

Compositions and Methods for Suppressing MSUT2

#549
20230233476
2023-07-27

NANOPARTICLE PHARMACEUTICAL COMPOSITIONS WITH REDUCED NANOPARTICLE SIZE AND IMPROVED POLYDISPERSITY INDEX

#550
20230227820
2023-07-20

RNA INTERFERENCE-INDUCING NUCLEIC ACID COMPRISING 8-OXOGUANINE, MODIFIED NUCLEIC ACID BINDING TO MICRORNA COMPRISING 8-OXOGUANINE, AND USES THEREOF

#551
20230226096
2023-07-20

CIRCULAR RNA COMPOSITIONS AND METHODS

#552
20230226095
2023-07-20

METHODS AND COMPOSITIONS FOR TREATING CORONAVIRUS INFECTIOUS DISEASE

#553
20230226086
2023-07-20

Methods of altering bone growth by administration of Sost or Wise antagonist or agonist

#554
20230225972
2023-07-20

LIPOSOMAL COMPOSITION FOR PREVENTING OR EARLY TREATMENT OF PATHOGENIC INFECTION

#555
20230220389
2023-07-13

NUCLEIC ACID MOLECULE TARGETING MITF GENE AND USE THEREOF

#556
20230220386
2023-07-13

SIRNA CONJUGATE, DOUBLE-STRANDED SIRNA CONJUGATE, SALT THEREOF AND APPLICATION THEREOF

#557
20230218656
2023-07-13

POLYPEPTIDES DIRECTED AGAINST VIRAL INFECTION AND USES THEREOF

#558
20230210886
2023-07-06

Pharmaceutical composition comprising organoid and anti-inflammatory agent for preventing or treating inflammatory bowel disease

#559
20230203500
2023-06-29

GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS

#560
20230203494
2023-06-29

AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME

#561
20230203491
2023-06-29

DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR TREATING COVID-19 CONTAINING SAME

#562
20230201363
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#563
20230201362
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#564
20230201245
2023-06-29

COMPOSITIONS AND METHODS FOR TREATING VIRUS INFECTION

#565
20230201244
2023-06-29

COMPOSITIONS AND METHODS FOR PREVENTING AND/OR TREATING MICROBIAL INFECTIONS

#566
20230201242
2023-06-29

RIG-I AGONISTS AND METHODS USING SAME

#567
20230193262
2023-06-22

Nucleic acid molecules capable of modulating target gene expression and uses thereof

#568
20230193258
2023-06-22

METHODS AND COMPOSITIONS FOR THE TREATMENT OF CANCER OR OTHER DISEASES

#569
20230192857
2023-06-22

INHIBITION OF CYTOKINE-INDUCED SH2 PROTEIN IN NK CELLS

#570
20230190785
2023-06-22

COMPOSITIONS AND METHODS FOR SILENCING DNAJC15 GENE EXPRESSION

#571
20230181682
2023-06-15

Compositions and methods for dengue virus chimeric constructions in vaccines

#572
20230181621
2023-06-15

ASPARAGINE SYNTHETASE INHIBITORS AND USES THEREOF

#573
20230181524
2023-06-15

PHARMACEUTICAL COMBINATION AND USE THEREOF

#574
20230181489
2023-06-15

COMBINATION THERAPIES TARGETING MITOCHONDRIAL BIOGENESIS FOR CANCER THERAPY

#575
20230174981
2023-06-08

HETERONUCLEIC ACID CONTAINING MORPHOLINO NUCLEIC ACID

#576
20230174980
2023-06-08

CHANNEL MODULATORS

#577
20230172963
2023-06-08

Methods of treating metabolic disorders and cardiovascular disease with inhibin subunit beta E (INHBE) inhibitors

#578
20230159933
2023-05-25

COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION

#579
20230159657
2023-05-25

Anti-tissue factor antibodies, antibody-drug conjugates, and related methods

#580
20230158061
2023-05-25

Nanotherapy Targeting RHAMM-Positive Tumors

#581
20230158060
2023-05-25

Inhibitors of C5a for the Treatment of Corona Virus Infection

#582
20230157956
2023-05-25

Oral Drug Delivery System and Method for Fabricating Thereof

#583
20230151365
2023-05-18

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#584
20230149316
2023-05-18

EDIBLE PLANT-DERIVED MICROVESICLE COMPOSITIONS FOR DIAGNOSIS AND TREATMENT OF DISEASE

#585
20230144623
2023-05-11

SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY

#586
20230142529
2023-05-11

RNA FORMULATIONS FOR HIGH VOLUME DISTRIBUTION

#587
20230141052
2023-05-11

Methods and compositions for genomic integration

#588
20230139944
2023-05-04

TARGETING ALPHA3BETA1 INTEGRIN FOR TREATMENT OF CANCER AND OTHER DISEASES

#589
20230139592
2023-05-04

SIRP-GAMMA TARGETED AGENTS FOR USE IN THE TREATMENT OF CANCER

#590
20230136613
2023-05-04

COMPOSITIONS AND METHODS FOR TREATING OR AMELIORATING INFECTIONS

#591
20230135432
2023-05-04

POLYMERIC NANOPARTICLES AND DERIVATIVES THEREOF FOR NUCLEIC ACID BINDING AND DELIVERY

#592
20230134572
2023-05-04

CHIMERIC RECEPTOR BINDING PROTEINS RESISTANT TO PROTEOLYTIC DEGRADATION

#593
20230133587
2023-05-04

Amino Acid Mediated Gene Delivery and Its Uses

#594
20230132645
2023-05-04

LIPID MEMBRANE STRUCTURE FOR DELIVERY INTO SIRNA CELL

#595
20230132582
2023-05-04

NOVEL USE OF ASPIRIN COMPOUND IN INCREASING NUCLEIC ACID EXPRESSION

#596
20230131243
2023-04-27

METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1

#597
20230126233
2023-04-27

LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#598
20230125671
2023-04-27

RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use

#599
20230124032
2023-04-20

Composition for preventing or treating keloids or hypertrophic scars

#600
20230123187
2023-04-20

METHODS AND COMPOSITIONS FOR TREATMENT OF ATHEROSCLEROSIS