20537 ⎘
Medicinal preparations containing organic active ingredients; Carbohydrates; Sugars; Derivatives thereof; Compounds having three or more nucleosides or nucleotides Double-stranded nucleic acids or oligonucleotides
COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#602METHODS FOR PREPARING NANOPARTICLE COMPOSITIONS CONTAINING HISTIDINE-LYSINE COPOLYMERS
#603Compositions and methods for delivery of RNA
#604RNAI INDUCED HUNTINGTIN GENE SUPPRESSION
#605COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#606NOVEL POLYINOSINIC - POLYCYTIDYLIC ACID COMPOSITIONS AND METHODS OF MAKING SAME
#607METHODS FOR CANCER TREATMENT
#608Transthyretin (TTR) iRNA compositions and methods of use thereof
#609Methods for treating hair loss disorders
#610USE OF CDK9 INHIBITORS TO REDUCE CARTILAGE DEGRADATION
#611TRIALKYL CATIONIC LIPIDS AND METHODS OF USE THEREOF
#612Nucleic acid and other compositions and methods for the modulation of cell membranes
#613GENE EDITING METHODS FOR TREATING SPINAL MUSCULAR ATROPHY
#614Compositions and methods for delivery of RNA
#615METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER
#616DELIVERY OF COMPOSITIONS COMPRISING CIRCULAR POLYRIBONUCLEOTIDES
#617Increasing gene expression
#618Nanoparticle compositions containing sugar functionalized nucleic acid carriers
#619NANOMETRIC PHARMACEUTICAL COMPOSITION IN THE FORM OF LIPOSOMES OR NANOEMULSION CONTAINING SPECIFIC SEQUENCES OF INTERFERENCE RNA
#620FUSOGENIC LIPOSOME-COATED POROUS SILICON NANOPARTICLES
#621RNAS FOR COMPLEMENT INHIBITION
#622STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#623COMBINATION THERAPY USING INHIBITORS OF HUMAN GROWTH AND DIFFERENTIATION FACTOR 15 (GDF-15) AND IMMUNE CHECKPOINT BLOCKERS
#624Methods of treating cancers having a BRCA1 and/or BRCA2 mutation(s)
#625Lipid compound as well as lipid carrier, nucleic acid lipid nanoparticle composition and pharmaceutical preparation containing same
#626COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSING OF METHYLATION-CONTROLLED J-PROTEIN (MCJ)
#627CLOSED-END DNA PRODUCTION WITH INVERTED TERMINAL REPEAT SEQUENCES
#628Compositions and methods for delivery of RNA
#629ANTISENSE OLIGONUCLEOTIDE TARGETING LINC00518 FOR TREATING MELANOMA
#630PRODUCTS AND COMPOSITIONS
#631Targeted therapy composition and its use for suppressing breast cancer cell proliferation, migration or invasion
#632NOVEL POLYINOSINIC - POLYCYTIDYLIC ACID COMPOSITIONS
#633DELIVERY COMPOSITIONS, AND METHODS OF MAKING AND USING SAME
#634METHODS AND COMPOSITIONS TO PREVENT AND TREAT INFLAMMATION AND ALLERGIC REACTIONS
#635ANTICANCER ADJUVANT AND PHARMACEUTICAL COMPOSITION FOR TREATING ANTICANCER-AGENT-RESISTANT CANCER, AND KIT COMPRISING SAME
#636USES OF BIOMARKERS FOR IMPROVING IMMUNOTHERAPY
#637METHODS OF TREATMENT OF CANCER DISEASE BY TARGETING AN EPIGENETIC FACTOR
#638METHODS AND COMPOSITIONS RELATING TO PROLONGED INFLAMMATORY INHIBITION AND/OR PROLONGED TREATMENT OF SPINAL PAIN BY CHIMERA DECOY
#639APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#640Methods and compositions for genomic integration
#641METHODS AND COMPOSITIONS FOR GENERATING TYPE 1 VESTIBULAR HAIR CELLS
#642Modulation Of Endoplasmic Reticulum Aminopeptidase 2 (ERAP2)-Mediated Immune Response
#643Methods and compositions for the specific inhibition of transthyretin (TTR) by double-stranded RNA
#644NORMALIZATION OF CULTURE OF CORNEAL ENDOTHELIAL CELLS
#645DELIVERY CARRIER INTO CELL
#646COMPOSITION FOR PREVENTING OR TREATING ISCHEMIA REPERFUSION INJURY COMPRISING NADPH OXIDASE 1 INHIBITOR AS ACTIVE INGREDIENT
#647COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#648A DELIVERY SYSTEM COMPRISING SILICON NANOPARTICLES
#649COMBINATION IMMUNOTHERAPIES FOR TREATMENT OF CANCER
#650Composition comprising PIC for treatment of cancer
#651COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#652COMPOSITIONS AND METHODS FOR HEMOGLOBIN PRODUCTION
#653Methods for treating hair loss disorders
#654Methods of treating skin cancer with Carboxypeptidase Vitellogenic Like (CPVL) inhibitors
#655INHIBITORS OF ADRENOMEDULLIN FOR THE TREATMENT OF ACUTE MYELOID LEUKEMIA BY ERADICATING LEUKEMIC STEM CELLS
#656THERAPEUTIC COMPOSITIONS CONTAINING BACTERIAL OUTER MEMBRANE VESICLES AND USES THEREOF
#657HSD17B13 VARIANTS AND USES THEREOF
#658MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#659APOLIPOPROTEIN B ANTAGONIST
#660Inhibitors of Cancer Biomarkers and Uses Thereof
#661Compounds and methods for reducing IFNAR1 expression
#662TREATMENT OF ABERRANT FIBROBLAST PROLIFERATION
#663METHOD FOR ALLEVIATING CANCER-INDUCED PAIN THROUGH CONTROL OF PAIN SIGNALS IN CENTRAL NERVOUS SYSTEM
#664EXTRAHEPATIC DELIVERY
#665Toxicity Management for Anti-Tumor Activity of CARs
#666EXOSOMES-BASED THERAPY FOR LIVER FIBROSIS AND OTHER DISEASES WITH FIBROSIS
#667RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#668Natural immunomodulator with antiviral activity
#669RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#670COMBINATION THERAPY FOR C3 INHIBITION
#671SBE APTAMERS FOR TREATING IL-17a RELATED DISEASES AND CONDITIONS
#672COMBINATION THERAPIES FOR THE TREATMENT OF CANCER
#673METHOD FOR TREATING CANCER
#674METHOD OF TREATING CANCER AND METHOD OF SENSITIZING CANCER CELLS TO THE ACTION OF CHEMOTHERAPEUTIC AGENTS VIA GROWTH HORMONE RECEPTOR ANTAGONISTS OR KNOCK DOWN
#675PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#676REGULATION OF RAN TRANSLATION BY PKR AND EIF2A-P PATHWAYS
#677NON-VIRAL VECTORS COMPRISING POLYPROPYLENEIMINE
#678Methods and compositions for synthesis of two-photon cleavable phosphoramidite molecules for oligonucleotide conjugation
#679ALDH3A2 INHIBITION AND FERROPTOSIS INDUCTION FOR CANCER THERAPY
#680METHODS FOR TREATING HEPATITIS B INFECTION
#681INHIBITION OF SMARCA2 FOR TREATMENT OF CANCER
#682METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#683ANTISENSE OLIGONUCLEOTIDE SEQUENCES FOR SILENCING THE HUMAN L1-MET TRANSCRIPT IN TUMORS
#684XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#685Hippo and dystrophin complex signaling in cardiomyocyte renewal
#686PHAGE COMPOSITIONS COMPRISING CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF
#687METHODS AND COMPOSITIONS FOR REPROGRAMMING CELLS
#688COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#689COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#690THYMIDINE KINASE GENE
#691Compositions and methods for delivery of RNA
#692COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF
#693Novel RNA Composition and Production Method for Use in iPS Cell Generation
#694NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#695Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof
#696METHOD FOR ASSESSING POSSIBILITY OF ONSET OR PROGRESSION OF CHRONIC KIDNEY ALLOGRAFT REJECTION AND CHRONIC KIDNEY DISEASE, TEST KIT, AND PHARMACEUTICAL COMPOSITION
#697Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof
#698Compositions and Methods for Simultaneously Modulating Expression of Genes
#699MODIFIED OLIGONUCLEOTIDES
#700ANTI-TIGIT ANTIBODIES AND METHODS OF USE THEREOF
#701Therapeutic double stranded RNA and methods for producing the same
#702COMBINED THERAPY FOR MUSCULAR DISEASES
#703Compositions and methods for transport across the blood brain barrier
#704Methods and compositions for treating endometriosis
#705Composition for preventing or treating fibrosis including an inhibitor of CDK17 expression or activity
#706COMPOSITIONS AND METHODS FOR TREATING CANCER
#707Methods For Directed Folding Assembly Or Dimerization Of Proteins By Templated Assembly Reactions
#708HLA CLASS I MOLECULES IN IN VITRO FERTILIZATION AND FURTHER MEDICAL IMPLICATIONS
#709Compositions and methods for delivery of RNA
#710Organic compositions to treat HSF1-related diseases
#711RNA interference mediated inhibition of prolyl hydroxylase domain 2 (PHD2) gene expression using short interfering nucleic acid (siNA)
#712Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof
#713SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF FOR CORONAVIRUS DISEASES
#714METHODS, COMPOSITIONS, AND VACCINES FOR TREATING A VIRUS INFECTION
#715Lipid nanoparticle compositions and methods for mRNA delivery
#716SYNTHETIC RIG-I-LIKE RECEPTOR AGONISTS
#717COMPOSITION FOR DETERMINATION OF CELL-MEDIATED IMMUNE RESPONSIVENESS
#718Method and carrier complexes for delivering molecules to cells
#719OLIGONUCLEOTIDES CONTAINING NUCLEOTIDE ANALOGS
#720FLUID DELIVERY SYSTEMS AND METHODS OF TREATMENT
#721Pharmaceutical compositions and related methods of delivery
#722Pharmaceutical compositions and related methods of delivery
#723Combination Treatments Of Cancer Comprising A TLR Agonist
#724NUCLEIC ACID COMPLEX
#725SYNERGISTIC IMMUNOSTIMULATION THROUGH THE DUAL ACTIVATION OF TLR3/9 WITH SPHERICAL NUCLEIC ACIDS
#726Treatment of inflammation with glucocorticoids and angiopoietin-like 7 (ANGPTL7) inhibitors
#727METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#728OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS
#729RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#730Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#731MicroRNA-33 inhibitors and use thereof in the treatment of pulmonary fibrosis
#732LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY
#733ADOPTIVE TRANSFER OF PLASMACYTOID DENDRITIC CELLS TO PREVENT OR TREAT HAIR LOSS
#734METHOD FOR TREATING MOOD DISORDERS
#735COMPOSITIONS AND METHODS USEFUL FOR EBOLA VIRUS INFECTION
#736p63 inactivation for the treatment of heart failure
#737GNAQ targeted dsRNA compositions and methods for inhibiting expression
#738BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#739TREATMENT OF TAUOPATHIES
#740USE OF REAGENT FOR DOWN-REGULATING CIRCULAR GENE EXPRESSION IN PREPARATION OF DRUGS FOR PREVENTING AND/OR TREATING PULMONARY FIBROSIS AND DRUG THEREOF
#741Products and methods for inhibition of expression of dynamin-1 variants
#742SiRNA, medical compositions, and methods for treating type ii diabetes using the same
#743Long Noncoding RNA Implicated in Cardiovascular Disease and Use Thereof
#744RNA vaccine against SARS-CoV-2 variants
#745TREATMENT METHODS USING ADENOVIRUS
#746Nucleic acids for inhibiting expression of TMPRSS6 and iron chelators
#747NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#748Nucleic acid-small diameter and liquid core nanoparticle complexed compositions
#749Materials And Methods Of Treating MHC-1-Opathy Risk Haplotypes
#750Pharmaceutical composition for treatment and prevention of chronic disease
#751AGENTS FOR THE TREATMENT OF DISEASES ASSOCIATED WITH UNDESIRED CELL PROLIFERATION
#752NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND CONJUGATE, PREPARATION METHOD THEREFOR AND USE THEREOF
#753Extended dicer substrate agents and methods for the specific inhibition of gene expression
#754Methods and Compositions for Selecting siRNA of Improved Functionality
#755Nucleic acid-polypeptide compositions and methods of inducing exon skipping
#756Methods of treating metabolic disorders and cardiovascular disease with Inhibin Subunit Beta E (INHBE) inhibitors
#757COMPOSITIONS FOR INTRATUMORAL ADMINISTRATION AND RELATED METHODS
#758EXTRACELLULAR VESICLES CONTAINING MIR-142-3P TO TREAT FIBROSING DISEASES
#759Using fatty acid synthase inhibitors to treat fibrosis
#760INHIBITION OF KMT2D FOR THE TREATMENT OF CANCER
#761RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF
#762COMBINATION OF HEPATITIS B VIRUS (HBV) VACCINES AND HBV-TARGETING RNAI
#763METHODS FOR THE TREATMENT OF ALPHA-1 ANTITRYPSIN DEFICIENCY (AATD)
#764SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#765GALNAC CLUSTER PHOSPHORAMIDITE AND TARGETED THERAPEUTIC NUCLEOSIDES
#766TARGETING CAPN9/CAPNS2 ACTIVITY AS A THERAPEUTIC STRATEGY FOR THE TREATMENT OF MYOFIBROBLAST DIFFERENTIATION AND ASSOCIATED PATHOLOGIES
#767RNA COMBINATIONS AND COMPOSITIONS WITH DECREASED IMMUNOSTIMULATORY PROPERTIES
#768THERAPEUTIC DRUG FOR DISEASES RELATED TO ENDOPLASMIC RETICULUM CELL DEATH IN CORNEAL ENDOTHELIUM
#769COMPOSITIONS AND METHODS FOR INHIBITING PCSK9
#770COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#771Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro
#772FLT3 ligand fusion proteins and methods of use
#773Tetragalnac and peptide containing conjugates and methods for delivery of oligonucleotides
#774Use of Thermostable RNA Polymerases to Produce RNAs Having Reduced Immunogenicity
#775METHODS OF CANCER TREATMENT BY DELIVERY OF siRNAs AGAINST BCLXL AND MCL1 USING A POLYPEPTIDE NANOPARTICLE
#776GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#777Compounds for Hepatitis B Treatment
#778COMBINED TRANSGENE AND INTRON-DERIVED MIRNA THERAPY FOR TREATMENT OF SCA1
#7792'-METHOXY SUBSTITUTED OLIGOMERIC COMPOUNDS AND COMPOSITIONS FOR USE IN GENE MODULATIONS
#780TREATMENT AND PREVENTION OF AGING RELATED-DISEASE AND/OR AGING BY THE INHIBITION OF SPHINGOLIPIDS
#781USE OF C3aR IN PREPARING DRUG FOR PREVENTING OR TREATING POLYCYSTIC KIDNEY DISEASE
#782HLA-H IN MEDICINE AND DIAGNOSTICS
#783HETEROCYCLIC COMPOUNDS FOR THE TREATMENT OF ARENAVIRUS INFECTION
#784DNA VACCINE AGAINST AMYLOID-BETA AND TAU
#785COMPOSITIONS AND METHODS FOR TREATING LONG COVID
#786COMPOUNDS AND METHODS FOR MODULATING CLN3 EXPRESSION
#787TREATMENT OF PULMONARY FIBROSIS USING INHIBITORS OF NEU1 SIALIDASE
#788TUNABLE LEUKOCYTE-BASED BIOMIMETIC NANOPARTICLES AND METHODS OF USE
#789METHOD AND COMPOSITION FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#790COMPOSITIONS AND METHODS FOR THE TREATMENT OF HYPERCHOLESTEROLEMIA
#791METHODS AND COMPOSITIONS FOR TREATING MALIGNANT TUMORS ASSOCIATED WITH KRAS MUTATION
#792COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#793NEUTRALIZING GRANZYME B FOR PROVIDING CARDIOPROTECTION IN A SUBJECT WHO EXPERIENCED A MYOCARDIAL INFARCTION
#794SELECTIVE LOCAL INHIBITION OF TNFR1-MEDIATED FUNCTIONS AT THE SITE OF ANTIGEN/ALLERGEN PRESENTATION
#795EXTENDED-RELEASE DRUG DELIVERY COMPOSITIONS
#796NANOMATERIALS CONTAINING CONSTRAINED LIPIDS AND USES THEREOF
#797COMPOSITIONS AND METHODS OF USING C/EBP ALPHA SARNA
#798HSD17B13 variants and uses thereof
#799BIODEGRADABLE CATIONIC POLYMERS AND USES THEREOF
#800Inhibition of cytokine-induced SH2 protein in NK cells
#801TARGETING PTPN22 IN CANCER THERAPY
#802COMPOSITIONS AND METHODS FOR DELIVERY OF AGENTS
#803CHIMERIC ANTIGENS FOR TREATING VIRAL INFECTION
#804Micro-RNAs and compositions comprising same for the treatment and diagnosis of serotonin-, adrenalin-, noradrenalin-, glutamate-, and corticotropin-releasing hormone- associated medical conditions
#805INCREASING ATOH1 LIFE TO DRIVE SENSORINEURAL HAIR CELL DIFFERENTIANTION
#806Anti-inflammatory treatment via inhibition of endothelial cell kinesin light chain 1, variant 1 (KLC1C)
#807COMPOSITIONS AND METHODS FOR ENHANCING INNATE IMMUNITY IN A SUBJECT FOR TREATMENT OF INFECTIONS AND CANCER AND OTHER ACUTE AND CHRONIC CONDITIONS OF THE EYE
#808METHOD OF TREATING AGE-RELATED MACULAR DEGENERATION
#809METASTASIS SPECIFIC SPLICE VARIANTS OF MENA AND USES THEREOF IN DIAGNOSIS, PROGNOSIS AND TREATMENT OF TUMORS
#810COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#811Methods and compositions related to RNA-targeted Rho small GTPase RND3/RhoE therapy
#812OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA
#813Compositions and methods for delivery of RNA
#814Biodegradable lipids for the delivery of active agents
#815TREATMENT AGENT FOR SEX HORMONE-INSENSITIVE GREB1-POSITIVE TUMORS
#816Surfactant peptide nanostructures and uses thereof in drug delivery
#817NANOVESICLES AND ITS USE FOR NUCLEIC ACID DELIVERY
#818NEURODEGENERATIVE DISEASE THERAPIES UTILIZING THE SKIN-BRAIN AXIS
#819Compositions and Methods for Monitoring, Diagnosis, Detection and Treatment of Cancer
#820APPLICATION OF CIRCULAR RNA IN PREPARING DRUG FOR TREATING SYSTEMIC LUPUS ERYTHEMATOSUS
#821TREATMENT OF HEART FAILURE IN HUMAN SUBJECTS
#822NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#823ENGINEERED ITR SEQUENCES AND METHODS OF USE
#824Lipid formulated compositions and methods for inhibiting expression of serum amyloid a gene
#825Ionizable compounds and compositions and uses thereof
#826ANTICANCER COMBINATIONS
#82725-HYDROXYCHOLESTEROL (25HC), CRYAB AGGREGATION INHIBITOR, IS A NOVEL SENOLYTIC
#828THERAPEUTIC AGENT FOR CANCER
#829Compositions and methods for monitoring, diagnosis, prognosis, detection, and treatment of cancer
#830RNAi Inhibition of Alpha-ENaC Expression
#831NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#832Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#833METHODS AND COMPOSITIONS FOR TREATING PULMONARY ARTERIAL HYPTERNSION
#834Compositions and methods for skin rejuvenation
#835SERPIN FAMILY F MEMBER 2 (SERPINF2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#836THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#837Compositions and methods for the delivery of nucleic acids
#838ENCAPSULATION OF MESSENGER RNA
#839METHODS AND COMPOSITIONS FOR TREATING MELANOMA
#840METHODS AND COMPOSITIONS OF SHORT SMALL HAIRPIN RNAS AND MICRORNAS FOR WOUND HEALING
#841METHOD FOR INHIBITING INFECTION AND ACTIVATION OF VIRUS
#842MODULATORS OF TELOMERE DISEASE
#843Sequence specific antimicrobials
#844Sequence specific antimicrobials
#845Sequence specific antimicrobials
#846Therapeutic pharmaceutical composition for cancer including miRNA
#847COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#848DUAL TARGETING siRNA AGENTS
#849DENDRITIC CELL IMMUNOTHERAPY
#850Bruton's Tyrosine Kinase as Anti-Cancer Drug Target
#851CROSS-LINKED POLYMER MODIFIED NANOPARTICLES
#852Treatment of amyotrophic lateral sclerosis (ALS)
#853ORAL DELIVERY OF OLIGONUCLEOTIDES
#854METHODS AND COMPOSITIONS OF MiR-10 MIMICS AND TARGETS THEREOF
#855METHODS FOR THE TREATMENT AND PROGNOSIS OF CANCER
#856SIRT1-SARNA COMPOSITIONS AND METHODS OF USE
#857OLIGOMERIC NUCLEIC ACID MOLECULE, AND APPLICATION THEREOF IN AN ACUTE INTERMITTENT PORPHYRIA TREATMENT
#858Nanoparticle to target cancer
#859Methods and Compositions for Treating Cancer
#860HIGH DENSITY LIPOPROTEIN NANOPARTICLES AND RNA TEMPLATED LIPOPROTEIN PARTICLES FOR OCULAR THERAPY
#861RAAV-based compositions and methods
#862LIPIDS AND LIPID NANOPARTICLE FORMULATIONS FOR DELIVERY OF NUCLEIC ACIDS
#863Agent for use in the treatment of glioma
#864RNA vaccine against SARS-CoV-2 variants
#865Therapeutic pharmaceutical composition for cancer including miRNA
#866HIGH DENSITY LIPOPROTEIN BINDING PROTEIN (HDLBP/VIGILIN) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#867IMMUNOSTIMULATING COMPOSITION
#868METHODS AND COMPOSITIONS FOR TREATING CANCER
#869RNA interference mediated inhibition of gene expression using short interfering nucleic acids (siNA)
#870COMPOSITIONS AND METHODS FOR INHIBITING CANCER STEM CELLS
#871MICRONEEDLE ARRAYS FOR CANCER THERAPY APPLICATIONS
#872NOVEL THERAPEUTIC AGENT FOR GASTROINTESTINAL CANCER AND METHOD FOR SCREENING FOR THE SAME
#873NXTAR-derived oligonucleotides and uses thereof
#874COMBINATION THERAPIES FOR THE TREATMENT OF ALZHEIMER'S DISEASE AND RELATED DISORDERS
#875Compounds for detecting and treating
#876SELECTIVE FOXO INHIBITORS FOR TREATMENT OF DIABETES AND OTHER DISORDERS RELATED TO IMPAIRED PANCREATIC FUNCTION
#877METHODS FOR MODULATING CHEMOTHERAPEUTIC CYTOTOXICITY
#878ESOPHAGEAL STRICTURE SUPPRESSING AGENT
#879PEPTIDE-FUNCTIONALIZED BIODEGRADABLE POLYMERS FOR EFFICIENT DELIVERY OF VARIOUS RNAS
#880A DELIVERY SYSTEM COMPRISING SILICON-CONTAINING MATERIAL
#881HIPK INHIBITORS AND METHODS OF USE THEREOF
#882MicroRNA-198 as a tumor suppressor in ovarian cancer
#883Modified short interfering nucleic acid (siNA) molecules and uses thereof
#884ENGINEERED EXOSOMES FOR TARGETED DELIVERY
#885CRISPR/CAS-BASED BASE EDITING COMPOSITION FOR RESTORING DYSTROPHIN FUNCTION
#886Biodegradable lipids for the delivery of active agents
#887Biodegradable lipids for the delivery of active agents
#888Biodegradable lipids for the delivery of active agents
#889Pharmaceutical Composition for Treating Muscle Disease
#890AIM2 INHIBITORS AND USES THEREOF
#891COMBINATION THERAPIES BASED ON PD1 AND IL-17B INHIBITORS
#892IMMUNOTHERAPY FOR THE TREATMENT OF CANCER
#893Methods for treating or preventing ophthalmological conditions
#894Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use
#895BLOCK COPOLYMERS AND USES THEREOF
#896INFLAMMASOME-TARGETED RNA INTERFERENCE APPROACH TO TREATING KIDNEY INJURY AND DISEASE
#897PIP4Ks SUPPRESS INSULIN SIGNALING AND ENHANCE IMMUNE FUNCTION THROUGH A CATALYTIC-INDEPENDENT MECHANISM
#898PRR-Activating and MicroRNA-Inhibiting Molecules and Methods of Using Same
#899RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#900Extended dicer substrate agents and methods for the specific inhibition of gene expression