ClassID:

20537

A61K31/713 - page 3 - CPC Classification

Classification description:

Medicinal preparations containing organic active ingredients; Carbohydrates; Sugars; Derivatives thereof; Compounds having three or more nucleosides or nucleotides Double-stranded nucleic acids or oligonucleotides

Recent Application in this class:
#601
20230121944
2023-04-20

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#602
20230121879
2023-04-20

METHODS FOR PREPARING NANOPARTICLE COMPOSITIONS CONTAINING HISTIDINE-LYSINE COPOLYMERS

#603
20230121003
2023-04-20

Compositions and methods for delivery of RNA

#604
20230119344
2023-04-20

RNAI INDUCED HUNTINGTIN GENE SUPPRESSION

#605
20230118337
2023-04-20

COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

#606
20230116048
2023-04-13

NOVEL POLYINOSINIC - POLYCYTIDYLIC ACID COMPOSITIONS AND METHODS OF MAKING SAME

#607
20230113240
2023-04-13

METHODS FOR CANCER TREATMENT

#608
20230111813
2023-04-13

Transthyretin (TTR) iRNA compositions and methods of use thereof

#609
20230111697
2023-04-13

Methods for treating hair loss disorders

#610
20230109457
2023-04-06

USE OF CDK9 INHIBITORS TO REDUCE CARTILAGE DEGRADATION

#611
20230109183
2023-04-06

TRIALKYL CATIONIC LIPIDS AND METHODS OF USE THEREOF

#612
20230109020
2023-04-06

Nucleic acid and other compositions and methods for the modulation of cell membranes

#613
20230108687
2023-04-06

GENE EDITING METHODS FOR TREATING SPINAL MUSCULAR ATROPHY

#614
20230107137
2023-04-06

Compositions and methods for delivery of RNA

#615
20230104125
2023-04-06

METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER

#616
20230104113
2023-04-06

DELIVERY OF COMPOSITIONS COMPRISING CIRCULAR POLYRIBONUCLEOTIDES

#617
20230101807
2023-03-30

Increasing gene expression

#618
20230100837
2023-03-30

Nanoparticle compositions containing sugar functionalized nucleic acid carriers

#619
20230099345
2023-03-30

NANOMETRIC PHARMACEUTICAL COMPOSITION IN THE FORM OF LIPOSOMES OR NANOEMULSION CONTAINING SPECIFIC SEQUENCES OF INTERFERENCE RNA

#620
20230095861
2023-03-30

FUSOGENIC LIPOSOME-COATED POROUS SILICON NANOPARTICLES

#621
20230095695
2023-03-30

RNAS FOR COMPLEMENT INHIBITION

#622
20230093948
2023-03-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#623
20230093412
2023-03-23

COMBINATION THERAPY USING INHIBITORS OF HUMAN GROWTH AND DIFFERENTIATION FACTOR 15 (GDF-15) AND IMMUNE CHECKPOINT BLOCKERS

#624
20230093238
2023-03-23

Methods of treating cancers having a BRCA1 and/or BRCA2 mutation(s)

#625
20230093138
2023-03-23

Lipid compound as well as lipid carrier, nucleic acid lipid nanoparticle composition and pharmaceutical preparation containing same

#626
20230092615
2023-03-23

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSING OF METHYLATION-CONTROLLED J-PROTEIN (MCJ)

#627
20230091932
2023-03-23

CLOSED-END DNA PRODUCTION WITH INVERTED TERMINAL REPEAT SEQUENCES

#628
20230091673
2023-03-23

Compositions and methods for delivery of RNA

#629
20230090446
2023-03-23

ANTISENSE OLIGONUCLEOTIDE TARGETING LINC00518 FOR TREATING MELANOMA

#630
20230089915
2023-03-23

PRODUCTS AND COMPOSITIONS

#631
20230089224
2023-03-23

Targeted therapy composition and its use for suppressing breast cancer cell proliferation, migration or invasion

#632
20230085710
2023-03-23

NOVEL POLYINOSINIC - POLYCYTIDYLIC ACID COMPOSITIONS

#633
20230084820
2023-03-16

DELIVERY COMPOSITIONS, AND METHODS OF MAKING AND USING SAME

#634
20230081146
2023-03-16

METHODS AND COMPOSITIONS TO PREVENT AND TREAT INFLAMMATION AND ALLERGIC REACTIONS

#635
20230080252
2023-03-16

ANTICANCER ADJUVANT AND PHARMACEUTICAL COMPOSITION FOR TREATING ANTICANCER-AGENT-RESISTANT CANCER, AND KIT COMPRISING SAME

#636
20230075965
2023-03-09

USES OF BIOMARKERS FOR IMPROVING IMMUNOTHERAPY

#637
20230070181
2023-03-09

METHODS OF TREATMENT OF CANCER DISEASE BY TARGETING AN EPIGENETIC FACTOR

#638
20230069350
2023-03-02

METHODS AND COMPOSITIONS RELATING TO PROLONGED INFLAMMATORY INHIBITION AND/OR PROLONGED TREATMENT OF SPINAL PAIN BY CHIMERA DECOY

#639
20230068339
2023-03-02

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#640
20230067484
2023-03-02

Methods and compositions for genomic integration

#641
20230061456
2023-03-02

METHODS AND COMPOSITIONS FOR GENERATING TYPE 1 VESTIBULAR HAIR CELLS

#642
20230059929
2023-02-23

Modulation Of Endoplasmic Reticulum Aminopeptidase 2 (ERAP2)-Mediated Immune Response

#643
20230058834
2023-02-23

Methods and compositions for the specific inhibition of transthyretin (TTR) by double-stranded RNA

#644
20230057984
2023-02-23

NORMALIZATION OF CULTURE OF CORNEAL ENDOTHELIAL CELLS

#645
20230055665
2023-02-23

DELIVERY CARRIER INTO CELL

#646
20230055500
2023-02-23

COMPOSITION FOR PREVENTING OR TREATING ISCHEMIA REPERFUSION INJURY COMPRISING NADPH OXIDASE 1 INHIBITOR AS ACTIVE INGREDIENT

#647
20230053332
2023-02-23

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#648
20230052784
2023-02-16

A DELIVERY SYSTEM COMPRISING SILICON NANOPARTICLES

#649
20230051860
2023-02-16

COMBINATION IMMUNOTHERAPIES FOR TREATMENT OF CANCER

#650
20230051846
2023-02-16

Composition comprising PIC for treatment of cancer

#651
20230047754
2023-02-16

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#652
20230045199
2023-02-09

COMPOSITIONS AND METHODS FOR HEMOGLOBIN PRODUCTION

#653
20230043374
2023-02-09

Methods for treating hair loss disorders

#654
20230037524
2023-02-09

Methods of treating skin cancer with Carboxypeptidase Vitellogenic Like (CPVL) inhibitors

#655
20230037414
2023-02-09

INHIBITORS OF ADRENOMEDULLIN FOR THE TREATMENT OF ACUTE MYELOID LEUKEMIA BY ERADICATING LEUKEMIC STEM CELLS

#656
20230035004
2023-02-02

THERAPEUTIC COMPOSITIONS CONTAINING BACTERIAL OUTER MEMBRANE VESICLES AND USES THEREOF

#657
20230031669
2023-02-02

HSD17B13 VARIANTS AND USES THEREOF

#658
20230028937
2023-01-26

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#659
20230027604
2023-01-26

APOLIPOPROTEIN B ANTAGONIST

#660
20230026844
2023-01-26

Inhibitors of Cancer Biomarkers and Uses Thereof

#661
20230025910
2023-01-26

Compounds and methods for reducing IFNAR1 expression

#662
20230024933
2023-01-26

TREATMENT OF ABERRANT FIBROBLAST PROLIFERATION

#663
20230018392
2023-01-19

METHOD FOR ALLEVIATING CANCER-INDUCED PAIN THROUGH CONTROL OF PAIN SIGNALS IN CENTRAL NERVOUS SYSTEM

#664
20230016929
2023-01-19

EXTRAHEPATIC DELIVERY

#665
20230013642
2023-01-19

Toxicity Management for Anti-Tumor Activity of CARs

#666
20230013636
2023-01-19

EXOSOMES-BASED THERAPY FOR LIVER FIBROSIS AND OTHER DISEASES WITH FIBROSIS

#667
20230013224
2023-01-19

RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use

#668
20230012579
2023-01-19

Natural immunomodulator with antiviral activity

#669
20230010288
2023-01-12

RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES

#670
20230009757
2023-01-12

COMBINATION THERAPY FOR C3 INHIBITION

#671
20230009539
2023-01-12

SBE APTAMERS FOR TREATING IL-17a RELATED DISEASES AND CONDITIONS

#672
20230008508
2023-01-12

COMBINATION THERAPIES FOR THE TREATMENT OF CANCER

#673
20230003732
2023-01-05

METHOD FOR TREATING CANCER

#674
20230002775
2023-01-05

METHOD OF TREATING CANCER AND METHOD OF SENSITIZING CANCER CELLS TO THE ACTION OF CHEMOTHERAPEUTIC AGENTS VIA GROWTH HORMONE RECEPTOR ANTAGONISTS OR KNOCK DOWN

#675
20230002772
2023-01-05

PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#676
20230002753
2023-01-05

REGULATION OF RAN TRANSLATION BY PKR AND EIF2A-P PATHWAYS

#677
20230000990
2023-01-05

NON-VIRAL VECTORS COMPRISING POLYPROPYLENEIMINE

#678
20230000983
2023-01-05

Methods and compositions for synthesis of two-photon cleavable phosphoramidite molecules for oligonucleotide conjugation

#679
20230000896
2023-01-05

ALDH3A2 INHIBITION AND FERROPTOSIS INDUCTION FOR CANCER THERAPY

#680
20230000895
2023-01-05

METHODS FOR TREATING HEPATITIS B INFECTION

#681
20230000849
2023-01-05

INHIBITION OF SMARCA2 FOR TREATMENT OF CANCER

#682
20220411817
2022-12-29

METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION

#683
20220411803
2022-12-29

ANTISENSE OLIGONUCLEOTIDE SEQUENCES FOR SILENCING THE HUMAN L1-MET TRANSCRIPT IN TUMORS

#684
20220411801
2022-12-29

XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#685
20220411798
2022-12-29

Hippo and dystrophin complex signaling in cardiomyocyte renewal

#686
20220411782
2022-12-29

PHAGE COMPOSITIONS COMPRISING CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF

#687
20220403390
2022-12-22

METHODS AND COMPOSITIONS FOR REPROGRAMMING CELLS

#688
20220403382
2022-12-22

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#689
20220403381
2022-12-22

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#690
20220401581
2022-12-22

THYMIDINE KINASE GENE

#691
20220401571
2022-12-22

Compositions and methods for delivery of RNA

#692
20220401563
2022-12-22

COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF

#693
20220396778
2022-12-15

Novel RNA Composition and Production Method for Use in iPS Cell Generation

#694
20220395580
2022-12-15

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#695
20220395526
2022-12-15

Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof

#696
20220390465
2022-12-08

METHOD FOR ASSESSING POSSIBILITY OF ONSET OR PROGRESSION OF CHRONIC KIDNEY ALLOGRAFT REJECTION AND CHRONIC KIDNEY DISEASE, TEST KIT, AND PHARMACEUTICAL COMPOSITION

#697
20220389428
2022-12-08

Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof

#698
20220389423
2022-12-08

Compositions and Methods for Simultaneously Modulating Expression of Genes

#699
20220389419
2022-12-08

MODIFIED OLIGONUCLEOTIDES

#700
20220389095
2022-12-08

ANTI-TIGIT ANTIBODIES AND METHODS OF USE THEREOF

#701
20220389050
2022-12-08

Therapeutic double stranded RNA and methods for producing the same

#702
20220387624
2022-12-08

COMBINED THERAPY FOR MUSCULAR DISEASES

#703
20220387612
2022-12-08

Compositions and methods for transport across the blood brain barrier

#704
20220387475
2022-12-08

Methods and compositions for treating endometriosis

#705
20220387473
2022-12-08

Composition for preventing or treating fibrosis including an inhibitor of CDK17 expression or activity

#706
20220387472
2022-12-08

COMPOSITIONS AND METHODS FOR TREATING CANCER

#707
20220387471
2022-12-08

Methods For Directed Folding Assembly Or Dimerization Of Proteins By Templated Assembly Reactions

#708
20220380848
2022-12-01

HLA CLASS I MOLECULES IN IN VITRO FERTILIZATION AND FURTHER MEDICAL IMPLICATIONS

#709
20220380810
2022-12-01

Compositions and methods for delivery of RNA

#710
20220380775
2022-12-01

Organic compositions to treat HSF1-related diseases

#711
20220380772
2022-12-01

RNA interference mediated inhibition of prolyl hydroxylase domain 2 (PHD2) gene expression using short interfering nucleic acid (siNA)

#712
20220380771
2022-12-01

Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof

#713
20220380770
2022-12-01

SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF FOR CORONAVIRUS DISEASES

#714
20220380769
2022-12-01

METHODS, COMPOSITIONS, AND VACCINES FOR TREATING A VIRUS INFECTION

#715
20220378939
2022-12-01

Lipid nanoparticle compositions and methods for mRNA delivery

#716
20220378817
2022-12-01

SYNTHETIC RIG-I-LIKE RECEPTOR AGONISTS

#717
20220373538
2022-11-24

COMPOSITION FOR DETERMINATION OF CELL-MEDIATED IMMUNE RESPONSIVENESS

#718
20220372172
2022-11-24

Method and carrier complexes for delivering molecules to cells

#719
20220372063
2022-11-24

OLIGONUCLEOTIDES CONTAINING NUCLEOTIDE ANALOGS

#720
20220370716
2022-11-24

FLUID DELIVERY SYSTEMS AND METHODS OF TREATMENT

#721
20220370622
2022-11-24

Pharmaceutical compositions and related methods of delivery

#722
20220370621
2022-11-24

Pharmaceutical compositions and related methods of delivery

#723
20220370606
2022-11-24

Combination Treatments Of Cancer Comprising A TLR Agonist

#724
20220370491
2022-11-24

NUCLEIC ACID COMPLEX

#725
20220370490
2022-11-24

SYNERGISTIC IMMUNOSTIMULATION THROUGH THE DUAL ACTIVATION OF TLR3/9 WITH SPHERICAL NUCLEIC ACIDS

#726
20220370489
2022-11-24

Treatment of inflammation with glucocorticoids and angiopoietin-like 7 (ANGPTL7) inhibitors

#727
20220364110
2022-11-17

METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION

#728
20220364100
2022-11-17

OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS

#729
20220364097
2022-11-17

RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS

#730
20220364096
2022-11-17

Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof

#731
20220364083
2022-11-17

MicroRNA-33 inhibitors and use thereof in the treatment of pulmonary fibrosis

#732
20220362406
2022-11-17

LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY

#733
20220362292
2022-11-17

ADOPTIVE TRANSFER OF PLASMACYTOID DENDRITIC CELLS TO PREVENT OR TREAT HAIR LOSS

#734
20220362203
2022-11-17

METHOD FOR TREATING MOOD DISORDERS

#735
20220356476
2022-11-10

COMPOSITIONS AND METHODS USEFUL FOR EBOLA VIRUS INFECTION

#736
20220348921
2022-11-03

p63 inactivation for the treatment of heart failure

#737
20220348915
2022-11-03

GNAQ targeted dsRNA compositions and methods for inhibiting expression

#738
20220347302
2022-11-03

BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS

#739
20220339183
2022-10-27

TREATMENT OF TAUOPATHIES

#740
20220339182
2022-10-27

USE OF REAGENT FOR DOWN-REGULATING CIRCULAR GENE EXPRESSION IN PREPARATION OF DRUGS FOR PREVENTING AND/OR TREATING PULMONARY FIBROSIS AND DRUG THEREOF

#741
20220333115
2022-10-20

Products and methods for inhibition of expression of dynamin-1 variants

#742
20220333114
2022-10-20

SiRNA, medical compositions, and methods for treating type ii diabetes using the same

#743
20220333109
2022-10-20

Long Noncoding RNA Implicated in Cardiovascular Disease and Use Thereof

#744
20220331422
2022-10-20

RNA vaccine against SARS-CoV-2 variants

#745
20220331383
2022-10-20

TREATMENT METHODS USING ADENOVIRUS

#746
20220331351
2022-10-20

Nucleic acids for inhibiting expression of TMPRSS6 and iron chelators

#747
20220324984
2022-10-13

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#748
20220323604
2022-10-13

Nucleic acid-small diameter and liquid core nanoparticle complexed compositions

#749
20220323581
2022-10-13

Materials And Methods Of Treating MHC-1-Opathy Risk Haplotypes

#750
20220323481
2022-10-13

Pharmaceutical composition for treatment and prevention of chronic disease

#751
20220323478
2022-10-13

AGENTS FOR THE TREATMENT OF DISEASES ASSOCIATED WITH UNDESIRED CELL PROLIFERATION

#752
20220315929
2022-10-06

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND CONJUGATE, PREPARATION METHOD THEREFOR AND USE THEREOF

#753
20220315925
2022-10-06

Extended dicer substrate agents and methods for the specific inhibition of gene expression

#754
20220315922
2022-10-06

Methods and Compositions for Selecting siRNA of Improved Functionality

#755
20220313833
2022-10-06

Nucleic acid-polypeptide compositions and methods of inducing exon skipping

#756
20220313726
2022-10-06

Methods of treating metabolic disorders and cardiovascular disease with Inhibin Subunit Beta E (INHBE) inhibitors

#757
20220313724
2022-10-06

COMPOSITIONS FOR INTRATUMORAL ADMINISTRATION AND RELATED METHODS

#758
20220313723
2022-10-06

EXTRACELLULAR VESICLES CONTAINING MIR-142-3P TO TREAT FIBROSING DISEASES

#759
20220313654
2022-10-06

Using fatty acid synthase inhibitors to treat fibrosis

#760
20220307031
2022-09-29

INHIBITION OF KMT2D FOR THE TREATMENT OF CANCER

#761
20220307022
2022-09-29

RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF

#762
20220305117
2022-09-29

COMBINATION OF HEPATITIS B VIRUS (HBV) VACCINES AND HBV-TARGETING RNAI

#763
20220305046
2022-09-29

METHODS FOR THE TREATMENT OF ALPHA-1 ANTITRYPSIN DEFICIENCY (AATD)

#764
20220305045
2022-09-29

SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#765
20220298508
2022-09-22

GALNAC CLUSTER PHOSPHORAMIDITE AND TARGETED THERAPEUTIC NUCLEOSIDES

#766
20220296688
2022-09-22

TARGETING CAPN9/CAPNS2 ACTIVITY AS A THERAPEUTIC STRATEGY FOR THE TREATMENT OF MYOFIBROBLAST DIFFERENTIATION AND ASSOCIATED PATHOLOGIES

#767
20220296628
2022-09-22

RNA COMBINATIONS AND COMPOSITIONS WITH DECREASED IMMUNOSTIMULATORY PROPERTIES

#768
20220296580
2022-09-22

THERAPEUTIC DRUG FOR DISEASES RELATED TO ENDOPLASMIC RETICULUM CELL DEATH IN CORNEAL ENDOTHELIUM

#769
20220290156
2022-09-15

COMPOSITIONS AND METHODS FOR INHIBITING PCSK9

#770
20220290152
2022-09-15

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE

#771
20220290150
2022-09-15

Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro

#772
20220289803
2022-09-15

FLT3 ligand fusion proteins and methods of use

#773
20220289785
2022-09-15

Tetragalnac and peptide containing conjugates and methods for delivery of oligonucleotides

#774
20220288240
2022-09-15

Use of Thermostable RNA Polymerases to Produce RNAs Having Reduced Immunogenicity

#775
20220288228
2022-09-15

METHODS OF CANCER TREATMENT BY DELIVERY OF siRNAs AGAINST BCLXL AND MCL1 USING A POLYPEPTIDE NANOPARTICLE

#776
20220288141
2022-09-15

GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS

#777
20220288102
2022-09-15

Compounds for Hepatitis B Treatment

#778
20220288101
2022-09-15

COMBINED TRANSGENE AND INTRON-DERIVED MIRNA THERAPY FOR TREATMENT OF SCA1

#779
20220288100
2022-09-15

2'-METHOXY SUBSTITUTED OLIGOMERIC COMPOUNDS AND COMPOSITIONS FOR USE IN GENE MODULATIONS

#780
20220288004
2022-09-15

TREATMENT AND PREVENTION OF AGING RELATED-DISEASE AND/OR AGING BY THE INHIBITION OF SPHINGOLIPIDS

#781
20220287998
2022-09-15

USE OF C3aR IN PREPARING DRUG FOR PREVENTING OR TREATING POLYCYSTIC KIDNEY DISEASE

#782
20220282330
2022-09-08

HLA-H IN MEDICINE AND DIAGNOSTICS

#783
20220281825
2022-09-08

HETEROCYCLIC COMPOUNDS FOR THE TREATMENT OF ARENAVIRUS INFECTION

#784
20220280619
2022-09-08

DNA VACCINE AGAINST AMYLOID-BETA AND TAU

#785
20220280547
2022-09-08

COMPOSITIONS AND METHODS FOR TREATING LONG COVID

#786
20220280545
2022-09-08

COMPOUNDS AND METHODS FOR MODULATING CLN3 EXPRESSION

#787
20220280472
2022-09-08

TREATMENT OF PULMONARY FIBROSIS USING INHIBITORS OF NEU1 SIALIDASE

#788
20220280428
2022-09-08

TUNABLE LEUKOCYTE-BASED BIOMIMETIC NANOPARTICLES AND METHODS OF USE

#789
20220280424
2022-09-08

METHOD AND COMPOSITION FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS

#790
20220275375
2022-09-01

COMPOSITIONS AND METHODS FOR THE TREATMENT OF HYPERCHOLESTEROLEMIA

#791
20220275373
2022-09-01

METHODS AND COMPOSITIONS FOR TREATING MALIGNANT TUMORS ASSOCIATED WITH KRAS MUTATION

#792
20220275365
2022-09-01

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#793
20220275105
2022-09-01

NEUTRALIZING GRANZYME B FOR PROVIDING CARDIOPROTECTION IN A SUBJECT WHO EXPERIENCED A MYOCARDIAL INFARCTION

#794
20220273791
2022-09-01

SELECTIVE LOCAL INHIBITION OF TNFR1-MEDIATED FUNCTIONS AT THE SITE OF ANTIGEN/ALLERGEN PRESENTATION

#795
20220273674
2022-09-01

EXTENDED-RELEASE DRUG DELIVERY COMPOSITIONS

#796
20220273566
2022-09-01

NANOMATERIALS CONTAINING CONSTRAINED LIPIDS AND USES THEREOF

#797
20220267770
2022-08-25

COMPOSITIONS AND METHODS OF USING C/EBP ALPHA SARNA

#798
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2022-08-25

HSD17B13 variants and uses thereof

#799
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2022-08-25

BIODEGRADABLE CATIONIC POLYMERS AND USES THEREOF

#800
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2022-08-25

Inhibition of cytokine-induced SH2 protein in NK cells

#801
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2022-08-25

TARGETING PTPN22 IN CANCER THERAPY

#802
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2022-08-25

COMPOSITIONS AND METHODS FOR DELIVERY OF AGENTS

#803
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2022-08-25

CHIMERIC ANTIGENS FOR TREATING VIRAL INFECTION

#804
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2022-08-25

Micro-RNAs and compositions comprising same for the treatment and diagnosis of serotonin-, adrenalin-, noradrenalin-, glutamate-, and corticotropin-releasing hormone- associated medical conditions

#805
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2022-08-18

INCREASING ATOH1 LIFE TO DRIVE SENSORINEURAL HAIR CELL DIFFERENTIANTION

#806
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2022-08-18

Anti-inflammatory treatment via inhibition of endothelial cell kinesin light chain 1, variant 1 (KLC1C)

#807
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2022-08-18

COMPOSITIONS AND METHODS FOR ENHANCING INNATE IMMUNITY IN A SUBJECT FOR TREATMENT OF INFECTIONS AND CANCER AND OTHER ACUTE AND CHRONIC CONDITIONS OF THE EYE

#808
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2022-08-18

METHOD OF TREATING AGE-RELATED MACULAR DEGENERATION

#809
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2022-08-11

METASTASIS SPECIFIC SPLICE VARIANTS OF MENA AND USES THEREOF IN DIAGNOSIS, PROGNOSIS AND TREATMENT OF TUMORS

#810
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2022-08-11

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE

#811
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2022-08-11

Methods and compositions related to RNA-targeted Rho small GTPase RND3/RhoE therapy

#812
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2022-08-11

OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA

#813
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2022-08-11

Compositions and methods for delivery of RNA

#814
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2022-08-11

Biodegradable lipids for the delivery of active agents

#815
20220249538
2022-08-11

TREATMENT AGENT FOR SEX HORMONE-INSENSITIVE GREB1-POSITIVE TUMORS

#816
20220249392
2022-08-11

Surfactant peptide nanostructures and uses thereof in drug delivery

#817
20220249376
2022-08-11

NANOVESICLES AND ITS USE FOR NUCLEIC ACID DELIVERY

#818
20220244275
2022-08-04

NEURODEGENERATIVE DISEASE THERAPIES UTILIZING THE SKIN-BRAIN AXIS

#819
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2022-08-04

Compositions and Methods for Monitoring, Diagnosis, Detection and Treatment of Cancer

#820
20220243270
2022-08-04

APPLICATION OF CIRCULAR RNA IN PREPARING DRUG FOR TREATING SYSTEMIC LUPUS ERYTHEMATOSUS

#821
20220243204
2022-08-04

TREATMENT OF HEART FAILURE IN HUMAN SUBJECTS

#822
20220243202
2022-08-04

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL

#823
20220243201
2022-08-04

ENGINEERED ITR SEQUENCES AND METHODS OF USE

#824
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2022-08-04

Lipid formulated compositions and methods for inhibiting expression of serum amyloid a gene

#825
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2022-08-04

Ionizable compounds and compositions and uses thereof

#826
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2022-08-04

ANTICANCER COMBINATIONS

#827
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2022-08-04

25-HYDROXYCHOLESTEROL (25HC), CRYAB AGGREGATION INHIBITOR, IS A NOVEL SENOLYTIC

#828
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2022-08-04

THERAPEUTIC AGENT FOR CANCER

#829
20220235422
2022-07-28

Compositions and methods for monitoring, diagnosis, prognosis, detection, and treatment of cancer

#830
20220235361
2022-07-28

RNAi Inhibition of Alpha-ENaC Expression

#831
20220235359
2022-07-28

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#832
20220235358
2022-07-28

Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof

#833
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2022-07-28

METHODS AND COMPOSITIONS FOR TREATING PULMONARY ARTERIAL HYPTERNSION

#834
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Compositions and methods for skin rejuvenation

#835
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2022-07-21

SERPIN FAMILY F MEMBER 2 (SERPINF2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#836
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2022-07-21

THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#837
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2022-07-21

Compositions and methods for the delivery of nucleic acids

#838
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2022-07-21

ENCAPSULATION OF MESSENGER RNA

#839
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METHODS AND COMPOSITIONS FOR TREATING MELANOMA

#840
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2022-07-14

METHODS AND COMPOSITIONS OF SHORT SMALL HAIRPIN RNAS AND MICRORNAS FOR WOUND HEALING

#841
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2022-07-14

METHOD FOR INHIBITING INFECTION AND ACTIVATION OF VIRUS

#842
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2022-07-14

MODULATORS OF TELOMERE DISEASE

#843
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2022-07-14

Sequence specific antimicrobials

#844
20220218796
2022-07-14

Sequence specific antimicrobials

#845
20220218795
2022-07-14

Sequence specific antimicrobials

#846
20220218733
2022-07-14

Therapeutic pharmaceutical composition for cancer including miRNA

#847
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2022-07-07

COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#848
20220213475
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DUAL TARGETING siRNA AGENTS

#849
20220213440
2022-07-07

DENDRITIC CELL IMMUNOTHERAPY

#850
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2022-07-07

Bruton's Tyrosine Kinase as Anti-Cancer Drug Target

#851
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2022-07-07

CROSS-LINKED POLYMER MODIFIED NANOPARTICLES

#852
20220211744
2022-07-07

Treatment of amyotrophic lateral sclerosis (ALS)

#853
20220211743
2022-07-07

ORAL DELIVERY OF OLIGONUCLEOTIDES

#854
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2022-07-07

METHODS AND COMPOSITIONS OF MiR-10 MIMICS AND TARGETS THEREOF

#855
20220211741
2022-07-07

METHODS FOR THE TREATMENT AND PROGNOSIS OF CANCER

#856
20220211740
2022-07-07

SIRT1-SARNA COMPOSITIONS AND METHODS OF USE

#857
20220211739
2022-07-07

OLIGOMERIC NUCLEIC ACID MOLECULE, AND APPLICATION THEREOF IN AN ACUTE INTERMITTENT PORPHYRIA TREATMENT

#858
20220211738
2022-07-07

Nanoparticle to target cancer

#859
20220211706
2022-07-07

Methods and Compositions for Treating Cancer

#860
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2022-07-07

HIGH DENSITY LIPOPROTEIN NANOPARTICLES AND RNA TEMPLATED LIPOPROTEIN PARTICLES FOR OCULAR THERAPY

#861
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RAAV-based compositions and methods

#862
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2022-06-30

LIPIDS AND LIPID NANOPARTICLE FORMULATIONS FOR DELIVERY OF NUCLEIC ACIDS

#863
20220202936
2022-06-30

Agent for use in the treatment of glioma

#864
20220202930
2022-06-30

RNA vaccine against SARS-CoV-2 variants

#865
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2022-06-30

Therapeutic pharmaceutical composition for cancer including miRNA

#866
20220202847
2022-06-30

HIGH DENSITY LIPOPROTEIN BINDING PROTEIN (HDLBP/VIGILIN) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#867
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IMMUNOSTIMULATING COMPOSITION

#868
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2022-06-30

METHODS AND COMPOSITIONS FOR TREATING CANCER

#869
20220195433
2022-06-23

RNA interference mediated inhibition of gene expression using short interfering nucleic acids (siNA)

#870
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2022-06-23

COMPOSITIONS AND METHODS FOR INHIBITING CANCER STEM CELLS

#871
20220193386
2022-06-23

MICRONEEDLE ARRAYS FOR CANCER THERAPY APPLICATIONS

#872
20220193113
2022-06-23

NOVEL THERAPEUTIC AGENT FOR GASTROINTESTINAL CANCER AND METHOD FOR SCREENING FOR THE SAME

#873
20220193110
2022-06-23

NXTAR-derived oligonucleotides and uses thereof

#874
20220193087
2022-06-23

COMBINATION THERAPIES FOR THE TREATMENT OF ALZHEIMER'S DISEASE AND RELATED DISORDERS

#875
20220186225
2022-06-16

Compounds for detecting and treating

#876
20220185797
2022-06-16

SELECTIVE FOXO INHIBITORS FOR TREATMENT OF DIABETES AND OTHER DISORDERS RELATED TO IMPAIRED PANCREATIC FUNCTION

#877
20220184111
2022-06-16

METHODS FOR MODULATING CHEMOTHERAPEUTIC CYTOTOXICITY

#878
20220184110
2022-06-16

ESOPHAGEAL STRICTURE SUPPRESSING AGENT

#879
20220183990
2022-06-16

PEPTIDE-FUNCTIONALIZED BIODEGRADABLE POLYMERS FOR EFFICIENT DELIVERY OF VARIOUS RNAS

#880
20220183989
2022-06-16

A DELIVERY SYSTEM COMPRISING SILICON-CONTAINING MATERIAL

#881
20220177891
2022-06-09

HIPK INHIBITORS AND METHODS OF USE THEREOF

#882
20220177889
2022-06-09

MicroRNA-198 as a tumor suppressor in ovarian cancer

#883
20220177888
2022-06-09

Modified short interfering nucleic acid (siNA) molecules and uses thereof

#884
20220177881
2022-06-09

ENGINEERED EXOSOMES FOR TARGETED DELIVERY

#885
20220177879
2022-06-09

CRISPR/CAS-BASED BASE EDITING COMPOSITION FOR RESTORING DYSTROPHIN FUNCTION

#886
20220175930
2022-06-09

Biodegradable lipids for the delivery of active agents

#887
20220175929
2022-06-09

Biodegradable lipids for the delivery of active agents

#888
20220175928
2022-06-09

Biodegradable lipids for the delivery of active agents

#889
20220175817
2022-06-09

Pharmaceutical Composition for Treating Muscle Disease

#890
20220175816
2022-06-09

AIM2 INHIBITORS AND USES THEREOF

#891
20220175815
2022-06-09

COMBINATION THERAPIES BASED ON PD1 AND IL-17B INHIBITORS

#892
20220175814
2022-06-09

IMMUNOTHERAPY FOR THE TREATMENT OF CANCER

#893
20220175813
2022-06-09

Methods for treating or preventing ophthalmological conditions

#894
20220170015
2022-06-02

Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use

#895
20220168448
2022-06-02

BLOCK COPOLYMERS AND USES THEREOF

#896
20220168444
2022-06-02

INFLAMMASOME-TARGETED RNA INTERFERENCE APPROACH TO TREATING KIDNEY INJURY AND DISEASE

#897
20220168402
2022-06-02

PIP4Ks SUPPRESS INSULIN SIGNALING AND ENHANCE IMMUNE FUNCTION THROUGH A CATALYTIC-INDEPENDENT MECHANISM

#898
20220168331
2022-06-02

PRR-Activating and MicroRNA-Inhibiting Molecules and Methods of Using Same

#899
20220162614
2022-05-26

RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS

#900
20220162608
2022-05-26

Extended dicer substrate agents and methods for the specific inhibition of gene expression