109047 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof General methods applicable to biologically active non-coding nucleic acids
Cas protein and use thereof in detection
#2INDUCIBLE PROMOTERS
#3OLIGONUCLEOTIDES
#4TYPE II CAS PROTEIN, CRISPR-CAS SYSTEM AND USES THEREOF
#5CELL THERAPY FOR ALZHEIMER'S DISEASE
#6COMPOSITIONS AND METHODS FOR EMR2 MODIFICATION
#7THERAPEUTIC AGENT, PROGRESSION INHIBITOR, AND PREVENTIVE AGENT FOR NEURODEGENERATIVE DISORDERS CHARACTERIZED BY AGGREGATION OF TDP43, TDP35, OR TDP25
#8MUTANTS FOR HAPLOID INDUCTION
#9METHODS AND COMPOSITIONS FOR HOMOLOGY DIRECTED REPAIR OF DOUBLE STRAND BREAKS IN PLANT CELL GENOMES
#10METHOD FOR USING GUIDE RNAS WITH CHEMICAL MODIFICATIONS
#11METHODS AND COMPOSITIONS FOR TREATING ALPHA-1 ANTITRYPSIN DEFICIENCY
#12COMPOSITIONS AND METHODS FOR GENOME EDITING
#13NANOS KNOCK-OUT THAT ABLATES GERMLINE CELLS
#14COMPOSITIONS AND METHODS FOR INCREASING PHYTOPHTHORA CROWN ROT RESISTANCE
#15Compositions and Methods for Targeted Delivery of CRISPR-CAS Effector Polypeptides and Transgenes
#16Fusion Geminin Protein
#17COMPOSITIONS AND METHODS COMPRISING PROGRAMMABLE SNRNAS FOR RNA EDITING
#18REPROGRAMABLE TNPB POLYPEPTIDES AND USE THEREOF
#19MICROFLUIDIC PLATFORM FOR THE STUDY OF MOLECULAR AND/OR CELLULAR INTERACTIONS
#20Compositions And Methods For Increasing Resistance To Nematodes In Plants
#21Polynucleotides, Compositions, and Methods for Genome Editing
#22MATERIALS AND METHODS FOR REDOSING SUBJECTS RECEIVING GENE INSERTION THERAPEUTICS
#23METHODS AND COMPOSITIONS FOR TRANSGENE DELIVERY AND/OR RECONSTITUTING MICROGLIA
#24NOVEL RECEPTORS FOR TRANSCRIPTION REGULATION
#25Method of Erasing Abnormal Epigenetic Modification in Ovine iCHI Embryo and Use in Generating Gene-Edited Sheep
#26Engineered Integration Enzymes and Uses Thereof
#27TREATMENT OF CANCERS HAVING A DRUG-RESISTANT MESENCHYMAL CELL STATE
#28MODIFIED HEMATOPOIETIC STEM CELLS AND PROGENIES THEREOF
#29POMPE DISEASE MOUSE MODEL GENERATION, CHARACTERIZATION AND METHODS OF USE
#30COMPARATIVE ASSESSMENT OF NANOPARTICLE DELIVERY VEHICLES
#31COMPOSITIONS AND METHODS COMPRISING PLANTS WITH MODIFIED SEED COMPOSITION
#32ENGINEERED PROTEINS AND METHODS OF USE THEREOF
#33MODULATORY POLYNUCLEOTIDES
#34NUCLEIC ACIDS AND USES THEREOF
#35RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#36ERRalpha GENE KNOCKOUT ERYTHROID PROGENITOR CELLS AND METHODS OF ERYTHROID DIFFERENTIATION THEREOF
#37MYOSTATIN PROTEIN MUTANT AND PREPARATION METHOD THEREOF
#38SUPPLEMENTATION OF LIVER ENZYME EXPRESSION
#39SUPPLEMENTATION OF LIVER ENZYME EXPRESSION
#40SUPPLEMENTATION OF LIVER ENZYME EXPRESSION
#41GENE CORRECTION INDUCED NEURAL STEM CELLS USING HUNTINGTIN GENE-SPECIFIC GUIDE RNA, AND CELL THERAPEUTIC AGENT USING THE SAME
#42METHODS FOR DETERMINATION AND MONITORING OF XENOTRANSPLANT REJECTION BY MEASURING NUCLEIC ACIDS OR PROTEINS DERIVED FROM THE XENOTRANSPLANT
#43DECREASING GENE EXPRESSION FOR INCREASED PROTEIN CONTENT IN PLANTS
#44HIGH-THROUGHPUT COMBINATORIAL GENETIC MODIFICATION SYSTEM AND OPTIMIZED CAS9 ENZYME VARIANTS
#45COMPOSITIONS AND METHODS FOR TREATMENT OF HYPERCHOLESTEROLEMIA AND/OR CARDIOVASCULAR DISEASE
#46METHODS FOR REPROGRAMMING AND GENE EDITING CELLS
#47VECTOR FOR MULTI-GENE BASE EDITING, EDITING METHOD, AND USE
#48Optimized SPCAS9 Proteins for Efficient Genome Editing in Eukaryotic Cells
#49METHOD FOR LOADING DIMERIC CD24 INTO HEK293 CELL EXTRACELLULAR VESICLES WITH ADAM10 GENE KNOCKED OUT
#50UORF EDITING TO IMPROVE PLANT TRAITS
#51ROOT-MEDIATED UPTAKE OF GUIDE RNA FOR GENOMIC EDITING OF A PLANT
#52METHODS AND MEANS FOR TRANSGENERATIONAL GENOME EDITING IN PLANTS
#53METHODS AND COMPOSITIONS FOR DESIGNING AND SELECTING TINYRNAS TO MAXIMIZE TARGET CLEAVAGE
#54MODIFIED DOUBLE-STRANDED RNA AGENTS
#55METHOD OF PREPARING SELF-CIRCULARIZED RNA
#56CRISPR/CPF1 Systems and Methods
#57EPIGENETIC EDITING TOOL FOR TARGETING HEPATITIS B VIRUS GENE
#58REMOVAL OF ENDOGENOUS TCR CHAINS FOR ENHANCED TCR-BASED IMMUNOTHERAPIES
#59RNA AND DNA BASE EDITING VIA ENGINEERED ADAR RECRUITMENT
#60METHODS FOR SELECTING VARIANT GUIDE RNA AND PRIME EDITING GUIDE RNA SCAFFOLDS, GUIDE RNA AND PRIME EDITING GUIDE RNA COMPOSITIONS AND METHODS OF USING THE SAME
#61CRISPR ENZYMES AND SYSTEMS
#62Method to Rejuvenate Human Cells Through Transcriptional Reprogramming
#63METHOD AND DEVICE FOR PREDICTING PRIME EDITING EFFICIENCY OF VARIOUS PRIME EDITORS IN DIFFERENT CELL TYPES
#64METABOLIC SELECTION VIA THE SERINE BIOSYNTHESIS PATHWAY
#65CRISPR-RELATED METHODS AND COMPOSITIONS TARGETING CD70 EXPRESSION
#66COMPOSITIONS AND METHODS FOR GENOME EDITING
#67SUSTAINED TRANSGENE EXPRESSION OF MODIFIED ERT2 PEPTIDE-SUICIDE PROTEIN FUSION POLYPEPTIDES
#68MODULAR BACTERIOPHAGE T4 NANOPARTICLE PLATFORM ENABLES RAPID DESIGN OF DUAL COVID-19-FLU MUCOSAL VACCINES
#69SYSTEMS FOR PRODUCTION OF TRANSDUCING PARTICLES, METHODS, KITS, COMPOSITIONS AND USES THEREOF
#70ACTIVATION AND PROLIFERATION OF CYTOTOXIC LYMPHOCYTES
#71NOVEL GENOMIC SAFE HARBOR AND USE THEREOF
#72METHOD FOR EFFICIENT GENETIC TRANSFORMATION AND GENE EDITING OF BRASSICA CROP MEDIATED BY AGROBACTERIUM RHIZOGENES
#73Method of Inhibiting Durotaxis and/or Treating Fibrosis
#74COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED GENE TARGETING FOR THE TREATMENT OF GENETIC DISORDERS IN ADULT PATIENTS
#75METHOD FOR PRODUCING A COMPUTATIONAL REDUCTION VACCINE
#76METHODS FOR IDENTIFYING TREATMENT TARGETS BASED ON MULTIOMICS DATA
#77ENGINEERED GENETIC INCOMPATIBILITY IN PLANTS
#78Oral Delivery of Antisense Conjugates Targeting PCSK9
#79METHODS OF PHAGE GENE MANIPULATION AND PROFILING
#80BIOMATERIALS AND PROCESSES FOR IMMUNE SYNAPSE MODULATION OF HYPOIMMUNOGENICITY
#81METHODS FOR IMPROVING PRODUCTION OF BIOLOGICAL PRODUCTS BY REDUCING THE LEVEL OF ENDOGENOUS PROTEIN
#82DRUG FOR GENETIC MODIFICATION, DRUG DELIVERY METHOD, AND DRUG DELIVERY CARRIER
#83METHODS OF GENOME EDITING OF CELLS WITH MODIFIED DONOR TEMPLATES
#84GENETIC CONSTRUCTS FOR GENE EDITING
#85LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#86TRITICEAE PLANT WITH SUPER-FLOWERING ABILITY, AND ITS PRODUCTION AND EVALUATION METHOD
#87MODIFIED OLIGONUCLEOTIDES
#88COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#89Differential Knockout of An Allele of A Heterozygous Fibrinogen Alpha Chain (FGA) Gene
#90CRISPR/CAS9-BASED REPRESSORS FOR SILENCING GENE TARGETS IN VIVO AND METHODS OF USE
#91EPIGENETIC MODULATION OF GENOMIC TARGETS TO CONTROL EXPRESSION OF PWS-ASSOCIATED GENES
#92COMPOSITIONS FOR AND METHODS OF EDITING THE GENOME
#93CYTIDINE DEAMINASE VARIANTS FOR BASE EDITING
#94Synthetic Nanostructures Including Nucleic Acids and/or Other Entities
#95HIGH-THROUGHPUT IN VIVO DNA RECOMBINEERING
#96POD SHATTER TOLERANCE IN BRASSICA PLANTS
#97METHODS AND COMPOSITIONS FOR TARGETING SERINE DEHYDRATASE
#98COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#99SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#100RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#101METHOD FOR PREPARING ENHANCED CAR-T-CELLS BASED ON INTERFERING OR KNOCKING OUT HUMAN PCSK9 GENE AND APPLICATION THEREOF
#102ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#103METHODS FOR TREATING ALZHEIMER'S DISEASE
#104CONSTRUCTION METHOD AND USE OF Thy1-SNCA; Clu GENE KNOCKOUT MOUSE MODEL
#105ENGINEERED CYTIDINE DEAMINASES
#106CRISPR SYSTEMS
#107COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#108LIPID NANOPARTICLE AND PHARMACEUTICAL COMPOSITION
#109NUCLEIC ACID CONSTRUCTS FOR GENOME EDITING
#110TXNIP INHIBITION TO ENHANCE ADOPTIVE IMMUNOTHERAPY
#111Delivery of RNA to Different Cell Types
#112ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#113METHODS AND COMPOSITIONS FOR MODIFICATION OF PROTOSPACER ADJACENT MOTIF SPECIFICITY OF CAS12A
#114METHODS AND COMPOSITIONS FOR MODIFICATION OF PROTOSPACER ADJACENT MOTIF SPECIFICITY OF CAS12A
#115COMPOSITIONS AND METHODS FOR TREATING ALPHA-1 ANTITRYPSIN DEFICIENCY
#116Antisense Nucleic Acids for Use in the Treatment for LMNA Mutation Carriers
#117METHODS AND COMPOSITIONS FOR SELECTIVELY ELIMINATING CELLS OF INTEREST
#118PHARMACEUTICAL COMPOSITION THAT INHIBITS PRODUCTION OF HEPATITIS B VIRUS PROTEIN, PHARMACEUTICAL COMPOSITION FOR TREATING HEPATITIS B, AND SCREENING METHOD
#119OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#120COMPOSITIONS AND METHODS FOR TARGETING, EDITING, OR MODIFYING GENES
#121SALT TOLERANT PLANTS
#122METAL HOMEOSTASIS REGULATION
#123COMPOSITIONS AND METHODS FOR IMPROVED NK CELL THERAPIES
#124MATERIALS AND METHODS FOR MODIFYING EXPRESSION OF MYOSIN HEAVY CHAIN GENES
#125METHODS OF IMPROVING SYSTEMIC DISEASE OUTCOMES BY INHIBITION OF ZHX2
#126CAS EXONUCLEASE FUSION PROTEINS AND ASSOCIATED METHODS FOR EXCISION, INVERSION, AND SITE SPECIFIC INTEGRATION
#127CRISPR INTERFERENCE THERAPEUTICS FOR C9ORF72 REPEAT EXPANSION DISEASE
#128CRISPR HYBRID DNA/RNA POLYNUCLEOTIDES AND METHODS OF USE
#129Selective Antisense Compounds and Uses Thereof
#130COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
#131SPLIT PRIME EDITORS
#132SYSTEMS AND METHODS FOR IDENTIFYING DNA SEQUENCES REGULATING PATTERN OF EXPRESSION FOR GENES OF INTEREST
#133Viral Diagnostic using CRISPR RNA combinations and Cas13a enzyme
#134ANTIMICROBIAL PEPTIDES
#135GIBBERELLIC ACID AND THE FORMATION OF MALE REPRODUCTIVE STRUCTURES ON FEMALE CANNABIS PLANTS
#136BUILDING DESIGNER RNA NANO-STRUCTURES FOR SYNTHETIC BIOLOGY APPLICATIONS
#137Oligomeric Compounds Comprising Bicyclic Nucleotides and Uses Thereof
#138Novel CRISPR-Cas delta enzyme and system
#139GENE THAT CONTROLS PARTHENOCARPIC FRUIT FORMATION AND USES THEREOF
#140POLYNUCLEIC ACID MOLECULES TARGETING AGT AND USES THEREOF
#141NOVEL SMALL TYPE V RNA PROGRAMMABLE ENDONUCLEASE SYSTEMS
#142SYSTEMS AND METHODS FOR GENETIC MODULATION TO TREAT LIVER DISEASE
#143NANOPARTICLE FORMULATIONS FOR DELIVERY OF NUCLEIC ACID COMPLEXES
#144METHODS FOR ENRICHING NUCLEIC ACID TARGET SEQUENCES
#145CRISPR/Cas9-BASED BASE EDITING OF TUBEROUS SCLEROSIS COMPLEX 2 GENE IN MESENCHYMAL STEM CELLS
#146CALCIUM SALTED SPHERICAL NUCLEIC ACIDS
#147Ligand-Modified Oligonucleotides
#148METHODS AND COMPOSITIONS FOR TREATING CANCERS BY MODULATING THE EXPRESSION AND/OR ACTIVITY OF STUB1
#149METHODS AND COMPOSITIONS FOR DISRUPTING NRF2-KEAP1 PROTEIN INTERACTION BY ADAR MEDIATED RNA EDITING
#150GENE-MODIFYING ENDONUCLEASES
#151CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#152COMPOSITION AND METHOD FOR TREATMENT OF LCA10 USING RNA-GUIDED NUCLEASE
#153CISH GENE EDITING OF TUMOR INFILTRATING LYMPHOCYTES AND USES OF SAME IN IMMUNOTHERAPY
#154GENOME EDITING IN PLANTS USING CAS12A NUCLEASES
#155COMPOSITIONS AND METHODS FOR NUCLEIC ACID TRANSFER
#156ENGINEERED Cas12f PROTEIN
#157BASE EDITING-MEDIATED READTHROUGH OF PREMATURE TERMINATION CODONS (BERT)
#158CRISPR-BASED MODULAR TOOL FOR THE SPECIFIC INTRODUCTION OF EPIGENETIC MODIFICATIONS AT TARGET LOCI
#159COMPOSITIONS AND METHODS FOR TREATING CANCER BY INCREASING EXPRESSION OF OBSCN-AS1 LONG-NONCODING RNA
#160METHODS AND COMPOSITIONS FOR MODULATING APOLIPOPROTEIN (A) EXPRESSION
#161MODIFIED RHABDOVIRUS GLYCOPROTEINS AND USES THEREOF
#162CONTEXT-SPECIFIC ADENINE BASE EDITORS AND USES THEREOF
#163ENGINEERED CAS ENDONUCLEASE VARIANTS FOR IMPROVED GENOME EDITING
#164NOVEL METHOD
#165Controlling Yeast Populations with Inter-Domain Genetic Modification via Conjugation Mediated Genetic Transfer
#166ENGINEERED GLYCOPROTEIN POPULATION AND USES THEREOF
#167ENGINEERED GLYCOPROTEIN POPULATION AND USES THEREOF
#168IDENTIFICATION OF TISSUE-SPECIFIC EXTRAGENIC SAFE HARBORS FOR GENE THERAPY APPROACHES
#169ANTI-CLL-1 CHIMERIC ANTIGEN RECEPTORS, ENGINEERED CELLS AND RELATED METHODS
#170SCREENING METHODS FOR TARGETS FOR CANCER THERAPY
#171METHOD FOR PREDICTING POSSIBLE OFF-TARGETS IN GENE EDITING PROCESS
#172MODIFIED AAV CONSTRUCTS AND USES THEREOF
#173PLANT REGULATORY ELEMENTS AND USES THEREOF FOR AUTOEXCISION
#174SOYBEAN PLANT CHARACTERIZED BY HIGH DROUGHT RESISTANCE
#175TISSUE-CULTURE INDEPENDENT GENE EDITING OF CELLS BY A LONG-DISTANCE RNA TRANSPORT SYSTEM
#176Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#177ADAPTATIONS FOR HIGH EFFICIENCY AND ALTERED PAM USAGE WITH TN7-CRISPR-CAS TRANSPOSITION SYSTEMS
#178REPROGRAMMABLE ISRB NUCLEASES AND USES THEREOF
#179PRIME EDITOR VARIANTS, CONSTRUCTS, AND METHODS FOR ENHANCING PRIME EDITING EFFICIENCY AND PRECISION
#180COMPOSITIONS AND METHODS FOR EDITING A TRANSTHYRETIN GENE
#181THERAPEUTIC APPLICATIONS OF CRISPR TYPE V SYSTEMS
#182Targeting Neo Splice Sites and Cryptic Exons in the Treatment of Cancer
#183A CLINICAL ISOLATED AVIRULENT STRAIN PROTECTS AGAINST WILDTYPE VIRULENT CLOSTRIDIOIDES DIFFICILE INFECTION
#184METHOD FOR PROMOTING SEXUAL MATURATION OF FISH
#185Novel Mutations in Streptococcus Pyogenes CAS9 Discovered by Broad Scanning Mutagenesis Demonstrate Enhancement of DNA Cleavage Activity
#186FLEXIBLE RNA SCAFFOLDING FOR REPROGRAMMABLE COMBINATORIAL RNAi ADMINISTRATION
#187SYSTEMS AND METHODS FOR GENE INSERTIONS
#188COMPLEX AND USE THEREOF
#189GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF FUCHS ENDOTHELIAL CORNEAL DYSTROPHY
#190METHODS AND MATERIALS FOR TREATING OBESITY
#191EVOLVED CYTOSINE DEAMINASES AND METHODS OF EDITING DNA USING SAME
#192THERAPEUTIC CRISPR/CAS9 GENE EDITING APPROACHES TO THE C9ORF72 REPEAT EXPANSION MUTATION IN IPSCS
#193CRISPR-Cas Effector Polypeptides and Methods of Use Thereof
#194TARGETED INTEGRATION AT ALPHA-GLOBIN LOCUS IN HUMAN HEMATOPOIETIC STEM AND PROGENITOR CELLS
#195ADENO-ASSOCIATED VIRUS CAPSIDS
#196COMPOSITIONS FOR RESTORING MECP2 GENE FUNCTION AND METHODS OF USE THEREOF
#197COMPOSITIONS AND METHODS FOR THE MANAGEMENT AND TREATMENT OF PHENYLKETONURIA
#198COMPOSITIONS AND METHODS FOR MODULATING A GENOME IN T CELLS, INDUCED PLURIPOTENT STEM CELLS, AND RESPIRATORY EPITHELIAL CELLS
#199GENOME EDITING OF CELLS
#200CREATE HUANGLONGBING TOLERANCE BY SILENCING A CITRUS NEGATIVE IMMUNE REGULATOR
#201HERBICIDE RESISTANCE
#202COMPOSITIONS AND METHODS FOR MODIFYING GENOMES
#203EDITING OLIGONUCLEOTIDE
#204NUCLEIC ACID NANOSWITCH CONSTRUCTION METHODS
#205METHOD OF SYNTHESIS OF AN IONIZABLE CATIONIC LIPID
#206VECTORS AND METHODS FOR IN VIVO ANTIBODY PRODUCTION
#207METHOD
#208OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#209ERYTHROPARVOVIRUS WITH A MODIFIED GENOME FOR GENE THERAPY
#210CD38 COMPOSITIONS AND METHODS FOR IMMUNOTHERAPY
#211SYSTEMS AND METHODS FOR RNA-GUIDED DNA INTEGRATION
#212GENOME EDITING OF B CELLS
#213USE OF SOYBEAN GENE GLYMA.13G252100 IN REGULATING RESISTANCE OF SOYBEAN TO PHYTOPHTHORA
#214USE OF MIR528 IN PRODUCTION AND BREEDING OF GRAMINEOUS FORAGE GRASSES
#215REGULATION OF TYPE I IFN SIGNALING BY TARGETING A DECOY RECEPTOR
#216Engineering of CAS9 Variants That Possess Targeted Nuclease Activity When Paired with Short SGRNAS
#217GENETICALLY-MODIFIED PLURIPOTENT STEM CELLS AND DERIVED NATURAL KILLER CELLS AND METHODS FOR PRODUCING THE SAME
#218ERYTHROPARVOVIRUS WITH A MODIFIED CAPSID FOR GENE THERAPY
#219COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#220COMPOSITIONS AND METHODS FOR MEDIATING EPITOPE ENGINEERING
#221ISOLATION OF ANTI-INFLAMMATORY NEUTROPHIL OR MONOCYTE SUBSET AND USE IN TREATING CARDIOVASCULAR DISEASES
#222SINGLE pegRNA-MEDIATED LARGE INSERTIONS
#223CONFERRING CYTOPLASMIC MALE STERILITY
#224EPICARDIAL CELL REGENERATION PROMOTER AND METHOD FOR PROMOTING EPICARDIAL CELL REGENERATION
#225MODRNA-BASED CAS ENDONUCLEASE AND BASE EDITOR AND USES THEREOF
#226ISOLATED CAS13 PROTEINS, GENE EDITING SYSTEM BASED THEREON, AND USE THEREOF
#227COMPOSITIONS AND METHODS FOR PROMOTING HOMOLOGY DIRECTED REPAIR
#228HOMOLOGY INDEPENDENT TARGETED INTEGRATION FOR GENE EDITING
#229RNA BASE EDITING COMPOSITIONS, SYSTEMS, METHODS AND USES THEREOF
#230TARGETED DNA INTEGRATION WITH LENTIVIRAL VECTORS AND USES THEREOF
#231METHODS AND SYSTEMS FOR DETECTING A TARGET USING BRCAS12B AND GENETICALLY ENGINEERED VARIANTS THEREOF
#232METHOD FOR PRODUCING POTATO PLANT WITH SUPPRESSED BROWNING USING CRISPR/Cas9 SYSTEM
#233ENHANCED CELL-FREE BACTERIOPHAGE SYNTHESIS BY GENETIC MODULATION OF BACTERIAL TRANSCRIPTION/TRANSLATION MACHINERY (TXTL) MACHINERY
#234ENGINEERING B CELL-BASED PROTEIN FACTORIES TO TREAT SERIOUS DISEASES
#235COMPOSITIONS AND METHODS FOR TREATING CHRONIC PAIN AND FOR RETROGRADE TRANSDUCTION OF NEURONS
#236TRANSGENIC ANIMAL HAVING MODIFIED MYOSTATIN GENE
#237KNOCKOUT OF A MUTANT ALLELE OF AN ELANE GENE
#238NOVEL CRISPR-CAS NUCLEASES FROM METAGENOMES
#239METHODS AND COMPOSITIONS FOR RE-DOSING AAV USING ANTI-CD40 ANTAGONISTIC ANTIBODY TO SUPPRESS HOST ANTI-AAV ANTIBODY RESPONSE
#240Methods and Compositions for Genetically Modifying a Cell
#241CO-DELIVERY OF INHIBITORY NUCLEIC ACIDS AND GENOME EDITORS FOR TUMOR THERAPY
#242Compositions and Methods for Genomic Editing
#243SYNTHESIS AND STORAGE OF DNA HAVING ATTACHED NANOSTRUCTURE
#244Conditional male sterility in wheat
#245BCAT gene controlling drought tolerance of plant and uses thereof
#246TARGETED AUGMENTATION OF NUCLEAR GENE OUTPUT
#247GUIDE RNAS AND USES THEREOF
#248RESCUE OF RECOMBINANT ADENOVIRUSES BY CRISPR/CAS-MEDIATED IN VIVO TERMINAL RESOLUTION
#249Methods and compositions for endogenous exon splicing using dCas13-RBM25 fusions
#250CATIONIC SULFONAMIDE AMINO LIPIDS AND AMPHIPHILIC ZWITTERIONIC AMINO LIPIDS
#251UTILIZATION OF GENE TARGETING ANTIBODY FUSION PROTEINS TO PERFORM IN VIVO THERAPEUTIC GENE EDITING
#252RT EDITING COMPOSITIONS AND METHODS
#253THERAPEUTIC LAMA2 PAYLOAD FOR TREATMENT OF CONGENITAL MUSCULAR DYSTROPHY
#254CHIMERIC ANTIGEN RECEPTOR COMPOSITIONS AND USES
#255GENE EDITING OF GBA1 IN STEM CELLS AND METHOD OF USE OF CELLS DIFFERENTIATED THEREFROM
#256TARGETED GENE INTEGRATION IN PLANTS
#257METHOD OF TREATING, AMELIORATING AND/OR PREVENTING POLYCYSTIC KIDNEY DISEASE
#258COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH siRNAS TARGETING TBX3
#259NOVEL SITES FOR SAFE GENOMIC INTEGRATION AND METHODS OF USE THEREOF
#260Guide RNA Constructs for Therapeutic Gene Editing
#261CYTOSINE DEAMINASE AND USE THEREOF IN BASE EDITING
#262LIPID NANOPARTICLES FOR GENE EDITING SYSTEMS
#263PRIMORDIAL GERM CELLS
#264DETERMINISTIC MECHANOPORATION FOR CELL ENGINEERING
#265DUAL VECTOR SELF-INACTIVATING CRISPR/CAS9 SYSTEM
#266Methods and Compositions for Inhibiting Viral Infection
#267RNA-GUIDED DNA TRANSPOSITION
#268METHODS FOR NOMINATION OF NUCLEASE ON-/OFF-TARGET EDITING LOCATIONS, DESIGNATED "CTL-seq" (CRISPR Tag Linear-seq)
#269REVERSIR TM COMPOUNDS
#270PEPTIDES AND NANOPARTICLES FOR INTRACELLULAR DELIVERY OF GENOME-EDITING MOLECULES
#271DNA REVERTASE
#272P-ETHOXY NUCLEIC ACIDS FOR LIPOSOMAL FORMULATION
#273METHODS AND COMPOSITIONS FOR TRANS-SPLICING UTILIZING SMALL NUCLEAR RNAS AND SMALL NUCLEOLAR RNAS
#274TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING
#275COMPOSITIONS, METHODS, AND SYSTEMS FOR DNA MODIFICATION
#276SERINE RECOMBINASE SYSTEMS FOR SITE-SPECIFIC GENE EDITING
#277Genes From Spinacia Tetrandra Encoding a Protein Providing Resistance Against Peronospora Farinosa and Spinach Plants Comprising These Genes
#278COMPOSITIONS AND METHODS FOR TRANSIENT GENE THERAPY WITH ENHANCED STABILITY
#279Oligonucleotides
#280CLASS 2 TYPE V CRISPR-CAS PRIME EDITING
#281METHODS AND COMPOSITIONS FOR USING PLASMA CELL DEPLETING AGENTS AND/OR B CELL DEPLETING AGENTS TO SUPPRESS HOST ANTI-AAV ANTIBODY RESPONSE AND ENABLE AAV TRANSDUCTION AND RE-DOSING
#282Inhibition of NHEJ, MMEJ, and 53BP1 Promotes High Levels of HDR
#283MULTI-TARGETED SINGLE ENTITY CONJUGATES
#284EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#285GENETICALLY ENGINEERED MESENCHYMAL STEM CELLS AND USES THEREOF
#286METHOD FOR TARGETED GENE INSERTION INTO IMMUNE CELLS
#287METHODS AND SYSTEMS FOR IDENTIFYING AND VALIDATING A GENE COMBINATION ASSOCIATED WITH A TRAIT AND USES THEREOF
#288USE OF APTAMERS IN PROTEOMICS
#289Use of Trinucleotide Repeat RNAs To Treat Cancer
#290METHODS AND COMPOSITIONS FOR THE MAKING AND USING OF GUIDE NUCLEIC ACIDS
#291GENE EDITING TO IMPROVE JOINT FUNCTION
#292COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING GPAM
#293COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#294Targeted CRISPR Delivery Platforms
#295PREPARATION AND ANTI-TUMOR APPLICATION OF GENE THERAPY VECTOR INTERFERING CKLF-LIKE MARVEL TRANSMEMBRANE DOMAIN-CONTAINING PROTEIN 6 (CMTM6) EXPRESSION
#296COMPOSITIONS AND METHODS FOR EFFICIENT IN VIVO DELIVERY
#297OPTIMIZED CAS PROTEIN AND USE THEREOF
#298HYPOIMMUNE BETA CELLS DIFFERENTIATED FROM PLURIPOTENT STEM CELLS AND RELATED USES AND METHODS
#299GENE EDITING SYSTEM FOR TREATING USHER SYNDROME
#300UNIVERSAL CELL AND METHOD FOR PREPARING SAME