109047 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof General methods applicable to biologically active non-coding nucleic acids
Production of reverse transcribed DNA (RT-DNA) using a retron reverse transcriptase from exogenous RNA
#302TARGET SYSTEM FOR HOMOLOGY-DIRECTED REPAIR AND GENE EDITING METHOD USING SAME
#303TUNING CASCADE ASSAY KINETICS VIA MOLECULAR DESIGN
#304NOVEL CRISPR ENZYMES AND SYSTEMS
#305RT-DNA Fidelity and Retron Genome Editing
#306METHODS AND COMPOSITIONS FOR SIMULTANEOUS EDITING OF BOTH STRANDS OF A TARGET DOUBLE-STRANDED NUCLEOTIDE SEQUENCE
#307RNA CAP ANALOGS AND METHODS OF USE
#308COMPOSITIONS INCLUDING IFNE AND USES THEREOF
#309COMPOSITIONS AND METHODS FOR TREATING A REFRACTORY OR RELAPSED CANCER OR A CHRONIC INFECTIOUS DISEASE
#310COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF
#311Compositions and Methods for TTR Gene Editing and Treating ATTR Amyloidosis
#312ENGINEERED CRISPR-CAS13F SYSTEM AND USES THEREOF
#313DEVELOPMENT OF RNA-TARGETED GENE EDITING TOOL
#314USE OF IRE1ALPHA-XBP1 SIGNALING PATHWAY BIOMARKERS FOR MODULATING IMMUNE RESPONSES
#315COMPOSITIONS COMPRISING A MUSCLE ACTIVE PROMOTER AND METHODS OF USING THE SAME
#316GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF
#317FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION
#318LIPID NANOPARTICLES
#319EFFICIENT SYNTHESIS AND ASSEMBLY METHOD FOR LARGE FRAGMENT DNA BASED ON PROGRAMMABLE NUCLEASE ARGONAUTE
#320Targeted CRISPR Delivery Platforms
#321MORPHOREGULATORS FOR REGENERATION OF MAIZE SOMATIC EMBRYOS
#322NOVEL CAS EFFECTOR PROTEINS, GENE EDITING SYSTEMS, AND USES THEREOF
#323GENETICALLY ENGINEERED T CELL FOR CELL THERAPY
#324LIPID NANOPARTICLES FOR TARGETED DELIVERY OF MRNA
#325A METHOD OF CELL ELECTROPORATION
#326Antisense Nucleic Acids
#327FULLY STABILIZED ASYMMETRIC SIRNA
#328SYSTEMS AND METHODS FOR GENETIC MODULATION TO TREAT OCULAR DISEASES
#329C2C9 NUCLEASE-BASED NOVEL GENOME EDITING SYSTEM AND USE THEREOF
#330ENGINEERED NUCLEASE AND USE THEREOF
#331Induction of IL-15/IL-15RA Expression in Immune Cells
#332COMPACT DRUG RESPONSIVE DOMAINS FOR REGULATION OF FUNCTION/ABUNDANCE AND DELIVERY OF POLYPEPTIDE PAYLOADS
#333ARTIFICIAL ANTIGEN-SPECIFIC IMMUNOREGULATORY T (AIRT) CELLS
#334ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#335FUSION PROTEINS
#336GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF GLYCOGEN STORAGE DISEASE TYPE 1B
#337CFTR-MODULATING COMPOSITIONS AND METHODS
#338COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#339COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#340FUSION PROTEINS AND USES THEREOF FOR PRECISION EDITING
#341CRISPR ENZYME MUTATIONS REDUCING OFF-TARGET EFFECTS
#342SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#343GENETICALLY ENGINEERED T CELLS WITH REGNASE-1 AND/OR TGFBRII DISRUPTION HAVE IMPROVED FUNCTIONALITY AND PERSISTENCE
#344Materials & Methods for Treatment of Macular Degeneration
#345MULTIPLEXED REPRESSION OF IMMUNOSUPPRESSIVE GENES
#346COMPOSITIONS FOR THE MODIFICATION OF THE HUMAN NRAS AND KRAS GENES
#347COMPOSITIONS AND METHODS FOR MODULATING ALPHA-SYNUCLEIN EXPRESSION
#348MODIFIED CRISPR-BASED GENE EDITING SYSTEM AND METHODS OF USE
#349USE OF CHEMICAL EPIGENETIC MODIFIERS TO MODULATE GENE EXPRESSION
#350METHODS AND MATERIALS FOR INHIBITING/PREVENTING THE TRAFFICKING OF MONOCYTES TO THE CENTRAL NERVOUS SYSTEM
#351RECOMBINANT ADENOVIRUS VACCINE FOR AFRICAN SWINE FEVER AND METHOD FOR CONSTRUCTING SAME
#352G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC
#353METHOD FOR PRODUCING PROLIFERATIVE MACROPHAGE-LIKE CELLS (pMAC)
#354TYPE I-B CRISPR-ASSOCIATED TRANSPOSASE SYSTEMS
#355COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#356Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#357Treatments of Disorders of Myelin
#358EPITOPE ENGINEERING OF CELL-SURFACE RECEPTORS
#359QUANTIFICATION OF ON-TARGET AND OFF-TARGET GENE EDITING ACTIVITY
#360SYSTEMS, METHODS, AND COMPOSITIONS FOR TARGETED GENE MANIPULATION AND USES THEREOF
#361Carrier for functional nucleic acid and protein introduction
#362COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#363COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#364COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#365COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#366COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#367COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#368COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#369COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#370ACTIVATION OF NONCODING HOST GENE LOCI
#371METHOD OF INTRODUCING A PLURALITY OF GENE DRIVES INTO A POPULATION
#372SYSTEMS AND METHODS OF NOVEL CRISPR-CAS PROTEINS FOR IN-VITRO APPLICATIONS
#373NUCLEIC ACID-GUIDED NICKASE FUSION PROTEINS
#374METHODS OF GENERATING A POPULATION OF NEURONS FROM HUMAN GLIAL PROGENITOR CELLS AND GENETIC CONSTRUCTS FOR CARRYING OUT SUCH METHODS
#375SUPPLEMENTATION OF LIVER ENZYME EXPRESSION
#376ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#377MEDICINE FOR DISEASE CAUSED BY FRAME-SHIFT MUTATION
#378GENE EDITING TO IMPROVE JOINT FUNCTION
#379MODIFIED IMMUNE EFFECTOR CELLS AND USES THEREOF
#380NUCLEIC ACID CONSTRUCT BASED ON CRE-LOXP AND CRISPR AND USE THEREOF
#381Applications of Streptococcus-derived Cas9 nucleases on minimal Adenine-rich PAM targets
#382MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
#383EFFECTOR PROTEINS AND METHODS OF USE
#384GUIDE OLIGONUCLEOTIDES FOR NUCLEIC ACID EDITING IN THE TREATMENT OF HYPERCHOLESTEROLEMIA
#385MUTANT CYTIDINE DEAMINASES WITH IMPROVED EDITING PRECISION
#386SYSTEMS AND METHODS FOR NUCLEIC ACID DETECTION
#387STREPTOCOCCUS PYOGENES-DERIVED CAS9 VARIANT
#388COMBINATION BCL11A ENHANCER EDITING
#389GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#390Method and Reagent Kit for Targeted Genomic Enrichment
#391Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#392METHODS AND COMPOSITIONS FOR TRICHOME REMOVAL
#393Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#394Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#395Compositions and Methods for Enhancing AAV Therapy and Decreasing Tropism of AAV to the Liver
#396Antisense Nucleic Acids
#397EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#398METHODS FOR IN VIVO DELIVERY AND DETECTION OF CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT SYSTEMS UTILIZING BACULOVIRUS VECTOR-MAGNETIC NANOPARTICLE COMPLEXES
#399T CELLS WITH IMPROVED FUNCTIONALITY
#400DISRUPTION OF THE SECRETION OF INSULIN-LIKE GROWTH FACTOR 2 FOR CANCER TREATMENT
#401METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES
#402ADENOSINE DEAMINASE BASE EDITORS AND METHODS FOR USE THEREOF
#403BASE EDITING AND CRISPR/CAS9 GENE EDITING STRATEGIES TO CORRECT CD3 SEVERE COMBINED IMMUNODEFICIENCY IN HEMATOPOIETIC STEM CELLS
#404METHOD FOR PRODUCING STERILIZED MALE INDIVIDUALS OF MARINE FISH, METHOD FOR PREVENTING REPRODUCTION OF MARINE FISH, AND STERILIZED MALE INDIVIDUALS OF MARINE FISH
#405ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF
#406COMPOSITIONS
#407ISOLATED NUCLEASE AND USE THEREOF
#408TRANSCRIPTION REGULATION SYSTEM BASED ON CRISPRI AND CRISPRA, AND ESTABLISHMENT METHOD THEREFOR AND USE THEREOF
#409DEPLETION OF CELLS BY CRISPR NUCLEASES
#410CELL-PENETRATING PEPTIDES FOR ANTISENSE DELIVERY
#411RECOMBINANT PRODUCTION OF PSILOCIN AND RELATED COMPOUNDS
#412METHOD FOR PRODUCING CELL HAVING DNA DELETION SPECIFIC TO ONE OF HOMOLOGOUS CHROMOSOMES
#413METHODS FOR GENOME EDITING
#414Oligonucleotides Comprising Modified Nucleosides
#415ENGINEERING CELLS FOR CELL-BASED THERAPIES, AND ASSOCIATED COMPOSITIONS AND METHODS
#416GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING STATHMIN 2 (STMN2) AND USES THEREOF
#417GENETICALLY MODIFIED CELLS FOR ALLOGENEIC CELL THERAPY TO REDUCE INSTANT BLOOD MEDIATED INFLAMMATORY REACTIONS
#418COMPOSITIONS AND METHODS FOR ENGINEERING STABLE TREGS
#419Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription
#420METHODS AND COMPOSITIONS FOR IMPROVING CROP YIELD TRAITS
#421Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#422HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#423OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#424Methylcytosine-Selective Deaminases and Uses Thereof
#425ENHANCED NUCLEIC ACID DETECTION USING CAS13 AND DESIGNED SECONDARY STRUCTURE
#426PROGRAMMABLE NUCLEASE-BASED ASSAY IMPROVEMENTS
#427GENOME EDITING WITH CRISPR/CAS NUCLEASES COMPRISING COLLATERAL ACTIVITY
#428MODULATORY POLYNUCLEOTIDES
#429SCHWANN CELL-SPECIFIC PROMOTER
#430METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#431COMPOSITIONS AND METHODS FOR CELL ENGINEERING FOR MEAT PRODUCTION
#432Gene Editing and Delivery of Myeloid Cells To Promote Wound Healing
#433THERAPEUTIC APPLICATIONS OF CPF1-BASED GENOME EDITING
#434CRYOGENICALLY ARRAYABLE STABLE TRANSFECTION
#435FUSION PROTEINS, COMPOSITIONS COMPRISING THE SAME, AND METHODS OF USE THEREOF
#436COMPOSITIONS AND METHODS FOR REDUCING COMPLEMENT ACTIVATION
#437TRIGGER NUCLEIC ACIDS AND RNA-BINDING PROTEINS FOR UPREGULATING GENE EXPRESSION
#438Exon skipping to treat Usher Syndrome
#439CRISPR-MEDIATED HUMAN GENOME EDITING WITH VECTORS
#440COMPOSITIONS AND METHODS FOR TREATMENT OF ANEUPLOID CANCERS
#441AMPLIFICATION ASSAYS USING CRISPR-CAS BASED DETECTION
#442Thermostable RNA Polymerase
#443METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#444OLIGONUCLEOTIDE MODULATORS ACTIVATING UTROPHIN EXPRESSION
#445COMPOSITIONS AND METHODS FOR TREATMENT OF TRANSTHYRETIN AMYLOIDOSIS
#446NOVEL CRISPR ENZYMES AND SYSTEMS
#447NOVEL CRISPR-CAS12I SYSTEMS AND USES THEREOF
#448GENE EDITING TO IMPROVE PANCREATIC BETA CELL YIELD IN DIRECTED DIFFERENTIATION OF HUMAN PLURIPOTENT STEM CELLS
#449Compositions And Methods For Regulating ZNF865
#450TARGETED COMPOSITIONS
#451CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING
#452EXTRACELLULAR VESICLES
#453IONIZABLE LIPIDS, LIPID NANOPARTICLES, AND USES THEREOF
#454COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#455IDENTIFICATION OF NANOPARTICLES FOR PREFERENTIAL TISSUE OR CELL TARGETING
#456Modified Oligonucleotides and Methods of Use
#457SYSTEMS, METHODS, AND COMPOSITIONS FOR SITE-SPECIFIC GENETIC ENGINEERING USING PROGRAMMABLE ADDITION VIA SITE-SPECIFIC TARGETING ELEMENTS (PASTE)
#458GUIDE RNA WITH CHEMICAL MODIFICATIONS
#459MICRORNA-33 INHIBITORS AND USE THEREOF IN THE TREATMENT OF PULMONARY FIBROSIS
#460METHODS AND SYSTEMS FOR CORRECTING MUTATIONS IN PRPH2
#461MITOCHONDRIAL BASE EDITORS AND METHODS FOR EDITING MITOCHONDRIAL DNA
#462Precise Excisions of Portions of Exon 44, 50, and 53 for Treatment of Duchenne Muscular Dystrophy
#463MODIFIED REGULATORY T CELLS AND METHODS OF USING THE SAME
#464GENETICALLY ENGINEERED CELLS HAVING ANTI-CD133 / ANTI-EGFR CHIMERIC ANTIGEN RECEPTORS, AND USES THEREOF
#465Expression Cassette for Production of High-Expression and High-Functionality Target Protein and Use Thereof
#466LODGING RESISTANCE IN ERAGROSTIS TEF
#467COMPOSITIONS AND METHODS FOR EFFICIENT IN VIVO DELIVERY
#468COMPOSITIONS AND METHODS FOR EFFICIENT IN VIVO DELIVERY
#469SYSTEMS FOR MODULATING DRUG METABOLISM BY CELLS, METHODS AND COMPOSITIONS THEREOF
#470STRATEGIES FOR DIRECT RECRUITMENT OF REPAIR TEMPLATES TO CRISPR NUCLEASES
#471PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES
#472SYSTEMS OF ENGINEERED RECEPTORS TARGETING PSMA AND CA9
#473METHODS OF EDITING NUCLEIC ACID SEQUENCES
#474OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION
#475GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF FRAGILE X SYNDROME
#476A METHOD FOR GENETIC MODIFICATION FOR HIGH GC CONTENT MICROORGANISMS
#477NUCLEIC ACID-GUIDED NUCLEASES
#478ELECTROPORATION ENHANCERS FOR CRISPR-CAS SYSTEMS
#479COMPOSITIONS AND METHODS COMPRISING PLANTS WITH MODIFIED SUGAR CONTENT
#480USE OF TAWOX FOR IMPROVING REGENERATION OF PLANT CELLS
#481METHODS FOR IMPROVING PROTEIN DELIVERY TO PLANT CELLS BY BIOLISTICS
#482COMPOSITIONS FOR INDUCING MODIFICATIONS OF TARGET ENDOGENOUS NUCLEIC ACID SEQUENCES IN NUCLEUSES OF EUKARYOTIC CELLS
#483METHODS AND AGENTS FOR INCREASING RBM3 EXPRESSION
#484Engineered Guide RNAs and Polynucleotides
#485AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF
#486ENDOGENOUS GENE REGULATION TO TREAT NEUROLOGICAL DISORDERS AND DISEASES
#487CD5 Modified Cells Comprising Chimeric Antigen Receptors (CARs) for Treatment of Solid Tumors
#488COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH
#489GENETICALLY MODIFIED RAT HAVING PKHD1L1 GENE WITH POINT MUTATION AND METHODS FOR ITS CONSTRUCTION, DETECTION AND USE
#490ANIMAL MODELS OF RECCURRENT HEPATOCELLULAR CARCINOMA AND USES THEREOF
#491METHOD FOR PRODUCING GENOME-EDITED CELLS UTILIZING HOMOLOGOUS RECOMBINATION
#492CLASS II, TYPE V CRISPR SYSTEMS
#493BIOACTIVE CONJUGATES FOR OLIGONUCLEOTIDE DELIVERY
#494MEDIA AND METHODS FOR MAKING AND MAINTAINING PORCINE PLURIPOTENT STEM CELLS
#495COMPOSITIONS AND METHODS FOR REDUCING PAIN AND INFLAMMATION THROUGH EPIGENETIC MODULATION
#496Co-Delivery of a Gene Editor Construct and a Donor Template
#497RNA EDITING VIA RECRUITMENT OF SPLICEOSOME COMPONENTS
#498ENGINEERED CAS12B EFFECTOR PROTEINS AND METHODS OF USE THEREOF
#499IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA
#500CELLS COMPRISING A SUPPRESSOR OF GENE EXPRESSION AND/OR A SYNTHETICPATHWAY ACTIVATOR AND/OR AN INDUCIBLE PAYLOAD
#501RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#502METHOD FOR NUCLEAR GENOME EDITING USING PLASTID SELECTABLE MARKERS
#503METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#504METHODS FOR DETERMINING INCREASED RISK OF CANCER DEVELOPMENT AND TREATING THE SAME
#505Precise Genome Editing Using Retrons
#506Engineered High Activity Omni-79 Nuclease Variants
#507NOVEL CRISPR-ASSOCIATED (CAS) PROTEIN
#508ANTISENSE NUCLEIC ACIDS
#509CANCER INTERVENTION BY TARGETING GENOTYPIC DIFFERENCES USING CRISPR-CAS3 MEDIATED DELETION-EDITING
#510A-REPEAT MINIGENE COMPOSITIONS FOR TARGETED REPRESSION OF SELECTED CHROMOSOMAL REGIONS AND METHODS OF USE THEREOF
#511METHODS FOR GENERATING GENETICALLY MODIFIED ANIMALS
#512SMALL NOVEL CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF
#513METHOD FOR EDITING BANANA GENES
#514MODIFIED DOUBLE-STRANDED RNA AGENTS
#515COMPOSITION FOR MODIFYING NUCLEIC ACID SEQUENCE, AND METHOD FOR MODIFYING TARGET SITE OF NUCLEIC ACID SEQUENCE
#516COMPOSITIONS AND METHODS FOR EFFICIENT IN VIVO DELIVERY
#517IMPROVED MODULAR PRIME EDITING WITH MODIFIED EFFECTORS AND TEMPLATES
#518CRISPR-MEDIATED TRANSGENE INSERTION IN NEONATAL CELLS
#519GENETICALLY MODIFIED CELLS AND METHODS OF MAKING AND USING SAME
#520DETECTING DISEASE-ASSOCIATED TARGET NUCLEIC ACIDS IN A MAMMAL AND TREATMENT THEREOF
#521METHODS FOR CREATING BILAYERS FOR USE WITH NANOPORE SENSORS
#522Conjugates of guide RNA-Cas protein complex for genome and epigenome editing
#523HIGH EFFICIENCY LARGE SCALE CHROMOSOMAL GENOME MANIPULATION
#524MIRROR-IMAGE SELECTION OF L-NUCLEIC ACID APTAMERS
#525NOVEL RNA BASE EDITING COMPOSITIONS, SYSTEMS, METHODS AND USES THEREOF
#526PACKAGING OLIGONUCLEOTIDES INTO VIRUS-LIKE PARTICLES
#527ADENOVIRUS DELIVERY SYSTEM FOR CANCER TREATMENT
#528STRATEGIES FOR KNOCK-INS AT C3 SAFE HARBOR SITES
#529Reduced Expression of Sarm1 For Use In Cell Therapy
#530PATHOGEN RESISTANCE IN PLANTS
#531METHODS AND COMPOSITIONS TARGETING NUCLEUS ACCUMBENS-ASSOCIATED PROTEIN-1 FOR TREATMENT OF AUTOIMMUNE DISORDERS AND CANCERS
#532Engineered Guide RNAs and Polynucleotides
#533METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES
#534NOVEL 5'-UNTRANSLATED REGION ELEMENT AND USE THEREOF
#535MODULATION OF THE CRISPR ROADBLOCK
#536METHODS OF EDITING WITH ENGINEERED CLASS 2 TYPE V CRISPR SYSTEMS
#537PROBES FOR DEPLETING ABUNDANT SMALL NONCODING RNA
#538ENGINEERED NUCLEASES, COMPOSITIONS, AND METHODS OF USE THEREOF
#539Engineered Cas protein and use thereof
#540RNA-Editing Compositions and Methods of Use
#541Sample splitting for multiplexed detection of nucleic acids without amplification
#542REGENERATION OR REJUVENATION OF TISSUES AND ORGANS
#543ENGINEERED AND CHIMERIC NUCLEASES
#544CPF1 PROTEIN AND ITS USE IN GENE EDITING
#545CLASS II, TYPE V CRISPR SYSTEMS
#546NRAS GENE KNOCKOUT FOR TREATMENT OF CANCER
#547METHODS RELATED TO MEGAKARYOCYTE-DERIVED EXTRACELLULAR VESICLES
#548Magnetic-Assisted Nanoparticle Delivery and Gene Editing Systems and Methods of Use
#549Compositions For and Methods of Improving Viral Vectors
#550NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#551METHOD
#552DEFINING SOURCE OF BITS IN TRIGGER FRAME FOR DISREGARD BITS AND RELEASING REDUNDANT BEAMFORMED BIT
#553EPIGENETIC TARGETS IN CLONAL HEMATOPOIESIS
#554Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#555SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
#556METHODS AND COMPOSITIONS FOR PRIME EDITING RNA
#557SMALL DNA CLOCKS COMPRISING A COMPOSITION FOR MEASURING OR PREDICTING THE DURATION OF CELLULAR EVENTS IN CELLS
#558SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#559CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR KNOCKING OUT C5
#560GENE EDITING TO TREAT MYELOPROLIFERATIVE NEOPLASMS
#561Method for the generation of genetically modified NK cells
#562Use of Inhibitors to Increase Efficiency of Crispr/CAS Insertions
#563METHODS AND COMPOSITIONS FOR GENOME EDITING
#564SYMRK PHOSPHORYLATION FOR ROOT NODULE ORGANOGENESIS
#565VECTORS AND METHODS FOR EFFICIENT CLONING AND HOMOLOGY DIRECTED REPAIR
#566MODIFIED DOUBLE-STRANDED RNA AGENTS
#567MODIFIED AAV CONSTRUCTS AND USES THEREOF
#568METHOD FOR ENHANCING THE SUSTAINED RELEASE ABILITY OF A NUCLEIC ACID DRUG
#569RNA-GUIDED TRANS-SPLICING OF RNA
#570IMPROVED PRIME EDITING SYSTEM EFFICIENCY WITH CIS-ACTING REGULATORY ELEMENTS
#571METHODS FOR UPREGULATING SHANK3 EXPRESSION
#572COMPOSITIONS AND METHODS FOR MULTIPLEX BASE EDITING IN HEMATOPOIETIC CELLS
#573METHOD FOR NARROWING EDITING WINDOW OF BASE EDITOR, BASE EDITOR, AND USE
#574CYTOKINE ASSOCIATED TUMOR INFILTRATING LYMPHOCYTES COMPOSITIONS AND METHODS
#575Tuning cascade assay kinetics via molecular design
#576MICRORNA-541-3P AS A THERAPEUTIC AGENT AS WELL AS ZNF101 AND CASZ1 AS THERAPEUTIC TARGETS TO LOWER PLASMA LDL-C, INCREASE PLASMA HDL-C, AND REDUCE ATHEROSCLEROSIS
#577EXPLOITING IL33 SECRETION AS A THERAPEUTIC TARGET IN CANCER
#578IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#579COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#580AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#581Chemically Modified Guide RNAs for CRISPR/CAS-Mediated Gene Correction
#582METHODS AND COMPOSITIONS FOR HIGH-THROUGHPUT PROTEIN DELIVERY, SCREENING, AND DETECTION
#583ENHANCED PROGRAMMABLE ADDITION VIA SITE-SPECIFIC TARGETING ELEMENTS SYSTEM USING A FUSION PROTEIN OF PRIME EDITOR PROTEIN AND PA01 INTEGRASE
#584Nucleic Acids and Methods for the Treatment of Pompe Disease
#585TARGET SEQUENCE SPECIFIC ALTERATION TECHNOLOGY USING NUCLEOTIDE TARGET RECOGNITION
#586METHODS FOR DELAYING CRISPR ACTION AND IMPROVING GENE DRIVE EFFECTIVENESS
#587COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#588GENE EDITING OF PCSK9 OR ANGPTL3 AND COMPOSITIONS AND METHODS OF USING SAME FOR TREATMENT OF DISEASE
#589CYTOKINE ASSOCIATED TUMOR INFILTRATING LYMPHOCYTES COMPOSITIONS AND METHODS
#590Synthesis of Oligonucleotides
#591Compositions And Methods For Promoting Gene Editing of CXCR4 Gene
#592COMPOSITIONS CONTAINING NUCLEIC ACID NANOPARTICLES AND PROCESSES RELATED TO ALTERATION OF THEIR PHYSIOCHEMICAL CHARACTERISTICS
#593Oligonucleotides
#594CELL POPULATIONS AND GENE EXPRESSION ASSOCIATED WITH IN VITRO BETA CELL DIFFERENTIATION
#595TREATMENT OF POLYCYTHEMIA VERA VIA CRISPR/AAV6 GENOME EDITING
#596LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#597GENOME EDITING OF GROWTH, DISEASE RESISTANCE/IMMUNITY AND CUTICLE COLOR IN CRUSTACEANS
#598PRIMATE DISEASE MODEL CONSTRUCTION METHOD BASED ON FAST GENE EDITION
#599COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#600CIRCULAR GUIDE RNAs FOR CRISPR/CAS EDITING SYSTEMS