109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING SICKLE CELL DISEASE
#3002INDUCTION OF REGULATORY B CELLS FOR THE TREATMENT OF IMMUNE-MEDIATED DISEASES
#3003Recombinant Adeno-Associated Virus Delivery of Exon 2-Targeted U7SNRNA Polynucleotide Constructs
#3004CRISPR/Cas-related methods and compositions for treating Leber's congenital amaurosis 10 (LCA10)
#3005METHODS FOR MODULATING SPLICING
#3006TREATMENT OF ABERRANT FIBROBLAST PROLIFERATION
#3007Nucleic acids for inhibiting expression of C3 in a cell
#3008NEUROFILAMENT LIGHT CHAIN (NFL) AS A BIOMARKER FOR TRANSTHYRETIN AMYLOIDOSIS POLYNEUROPATHY
#3009BLOOD-BRAIN BARRIER PERMEABLE HETERODUPLEX NUCLEIC ACID
#3010Modulation of huntingtin expression
#3011COMPOSITIONS AND METHODS FOR INSECT CONTROL
#3012NOVEL RNA THERAPEUTICS AND USES THEREOF
#3013Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#3014Methods for reactivating genes on the inactive X chromosome
#3015COMPOUNDS AND METHODS FOR MODULATING C90RF72
#3016COMPOSITIONS FOR DELIVERY OF ANTISENSE COMPOUNDS
#3017Nucleic acids for inhibiting expression of PROS1 in a cell
#3018NK CELL-BASED THERAPY
#3019INHIBITING THE RNA METHYLTRANSFERASE METTL3 OR ITS INTERACTION WITH EIF3H TO SUPPRESS ONCOGENE TRANSLATION AND TUMORIGENESIS
#3020Calcium Channel 3.2 Inhibitory Peptides and Uses Thereof
#3021EXTRACELLULAR VESICLES WITH ANTISENSE OLIGONUCLEOTIDES TARGETING KRAS
#3022EXTRAHEPATIC DELIVERY
#3023Signal-sensor polynucleotides for the alteration of cellular phenotypes
#3024EXOSOMES-BASED THERAPY FOR LIVER FIBROSIS AND OTHER DISEASES WITH FIBROSIS
#3025REGENERATING FUNCTIONS AND PHENOTYPES OF CONNECTIVE TISSUE THROUGH NPAS2 SUPPRESSION
#3026RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#3027RNAi Agents for Inhibiting Expression of Beta-ENaC, Compositions Thereof, and Methods of Use
#3028NUCLEOSIDE DERIVATIVE AND USE THEREOF
#3029TISSUE FOR USE AS ALLOGENEIC OR XENOGENEIC TRANSPLANT AND METHOD FOR ITS PRODUCTION
#3030RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#3031COMBINATION THERAPY FOR C3 INHIBITION
#3032METHOD FOR PROVIDING IMMUNE CELLS WITH ENHANCED FUNCTION
#3033LIGATION-BASED GENE EDITING USING CRISPR NICKASE
#3034Application of CAS protein, method for detecting target nucleic acid molecule and kit
#3035Compositions and methods for inhibiting gene expression of alpha-1 antitrypsin
#3036RNAi Agents for Inhibiting Expression of Mucin 5AC (MUC5AC), Compositions Thereof, and Methods of Use
#3037CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY
#3038METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#3039EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING CEBP/BETA
#3040Selective antisense compounds and uses thereof
#3041CRISPR/CAS-RELATED METHODS, COMPOSITIONS AND COMPONENTS
#3042Vitro Cleavage of DNA Using Argonaute
#3043SELECTIVE EXPANSION OF GENE-TARGETED CELLS
#3044Adeno-Associated Virus Vector Delivery of Microrna-29 to Treat Muscular Dystrophy
#3045Muscle targeting complexes and uses thereof for treating dystrophinopathies
#3046COMPOSITIONS AND METHODS FOR NUCLEIC ACID DELIVERY
#3047METHODS FOR TREATING HEPATITIS B INFECTION
#3048DUAL SUPRAMOLECULAR NANOPARTICLE VECTORS ENABLE CRISPR/CAS9-MEDIATED KNOCKIN OF RETINOSCHISIN 1 GENE-A POTENTIAL NON-VIRAL THERAPEUTIC SOLUTIONS FOR X-LINKED JUVENILE RETINOSCHISIS
#3049PROGRAMMABLE NUCLEASE COMPOSITIONS AND METHODS OF USE THEREOF
#3050PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF
#3051NUCLEIC ACID MOLECULES CONTAINING SPACERS AND METHODS OF USE THEREOF
#3052METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#3053CHIMERIC TRANSCRIPTION FACTOR VARIANTS WITH AUGMENTED SENSITIVITY TO DRUG LIGAND INDUCTION OF TRANSGENE EXPRESSION IN MAMMALIAN CELLS
#3054Hippo and dystrophin complex signaling in cardiomyocyte renewal
#3055Twist signaling inhibitor compositions and methods of using the same
#3056COMPOSITIONS AND METHODS FOR DECREASING TAU EXPRESSION
#3057ENGINEERED CELLS FOR CONTROLLED PRODUCTION
#3058RNA OLIGONUCLEOTIDES FOR PREVENTING AGGREGATION OF PROTEINS
#3059Compounds and methods for modulating UBE3A-ATS
#3060NUCLEIC ACID COMPOSITIONS
#3061METHODS OF PERFORMING RNA TEMPLATED GENOME EDITING
#3062METHOD OF TRANSACTIVATING A HOMOLOGOUS GENE OF A GENE OF INTEREST AND AN IN VITRO METHOD OF DIAGNOSING A DISEASE
#3063Control of plant pests using RNA molecules
#3064RNAI-MEDIATED PEST CONTROL
#3065Modulation of Angiopoietin-Like 3 Expression
#3066METHODS AND COMPOSITIONS FOR REPROGRAMMING CELLS
#3067THERAPEUTIC OLIGONUCLEOTIDE METHODS
#3068Oligonucleotide Progranulin Agonists
#3069MODULATING GENOMIC COMPLEXES
#3070Selective reduction of allelic variants
#3071COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#3072ENGINEERED CIRCULAR RNA CIRCMIR-29B AND USE THEREOF IN PREPARATION OF MEDICINE FOR TREATING MUSCLE ATROPHY
#3073METHODS AND COMPOSITIONS FOR MODULATING SPLICING
#3074COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#3075COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3076RNA Interactome of Polycomb Repressive Complex 1 (PRC1)
#3077MODIFIED iRNA AGENTS
#3078Closed process for expansion and gene editing of tumor infiltrating lymphocytes and uses of same in immunotherapy
#3079Closed process for expansion and gene editing of tumor infiltrating lymphocytes and uses of same in immunotherapy
#3080Trialkyne linking agents and methods of use
#3081COMPOSITIONALLY DEFINED PLASMID DNA/POLYCATION NANOPARTICLES AND METHODS FOR MAKING THE SAME
#3082COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF
#3083REFILLABLE DRUG DELIVERY DEVICES AND METHODS OF USE THEREOF
#3084RNA-guided nucleic acid modifying enzymes and methods of use thereof
#3085Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA
#3086METHOD FOR PRODUCING NUCLEIC ACID MOLECULE, BIOMATERIAL, AND METHOD FOR PRODUCING BIOMATERIAL
#3087RNAi Agents for Inhibiting Expression of Receptor for Advanced Glycation End-products, Compositions Thereof, and Methods of Use
#3088Novel RNA Composition and Production Method for Use in iPS Cell Generation
#3089Closed process for expansion and gene editing of tumor infiltrating lymphocytes and uses of same in immunotherapy
#3090CLOSED PROCESS FOR EXPANSION AND GENE EDITING OF TUMOR INFILTRATING LYMPHOCYTES AND USES OF SAME IN IMMUNOTHERAPY
#3091NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#3092TREATMENT OF COVID-19 LUNG INJURY USING UMBILICAL CORD PLASMA BASED COMPOSITIONS
#3093METHOD FOR ASSESSING POSSIBILITY OF ONSET OR PROGRESSION OF CHRONIC KIDNEY ALLOGRAFT REJECTION AND CHRONIC KIDNEY DISEASE, TEST KIT, AND PHARMACEUTICAL COMPOSITION
#3094SYSTEM AND METHOD FOR COMBATING INFECTIONS DUE TO PATHOGENS BELONGING TO PHYLUM PROTEOBACTERIA
#3095ANALYSIS OF NUCLEIC ACIDS ASSOCIATED WITH SINGLE CELLS USING NUCLEIC ACID BARCODES
#3096ANALYSIS OF NUCLEIC ACIDS ASSOCIATED WITH SINGLE CELLS USING NUCLEIC ACID BARCODES
#3097MATERIALS AND METHODS FOR THE TREATMENT OF DISORDERS ASSOCIATED WITH THE IRF2BPL GENE
#3098miRNA AS BIOMARKER FOR PARKINSON'S DISEASE AND DIAGNOSTIC KIT USING SAME
#3099Mbp_Argonaute proteins from prokaryotes and applications thereof
#3100Modified double-stranded RNA agents
#3101Compositions and Methods for Simultaneously Modulating Expression of Genes
#3102IONIZABLE CATIONIC LIPIDS FOR RNA DELIVERY
#3103RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS
#3104AGENTS FOR THE TREATMENT OF PATIENTS WITH NSCLC AND METHODS TO PREDICT RESPONSE
#3105MODIFIED OLIGONUCLEOTIDES
#3106Nucleic acid-guided nucleases
#3107CHIMERIC GENOME ENGINEERING MOLECULES AND METHODS
#3108Compositions and methods of treatment
#3109Compositions and Methods for Treating Cancer with Anti-ROR1 Immunotherapy
#3110Compositions and methods for transport across the blood brain barrier
#3111EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#3112CONJUGATES AND METHODS FOR TREATING LIVER FIBROSIS
#3113Treating and preventing infections
#3114TREATMENTS FOR CHARCOT-MARIE-TOOTH DISEASE
#3115Compositions and methods for organ specific delivery of nucleic acids
#3116METHOD FOR REDUCING THE EXPRESSION OF NKCC1 IN A SUBJECT
#3117METHODS AND COMPOSITIONS FOR MODIFYING ROOT ARCHITECTURE IN PLANTS
#3118Organic compositions to treat HSF1-related diseases
#3119TARGETING NONSENSE-MEDIATED DECAY TO ACTIVATE P53 PATHWAY FOR THE TREATMENT OF CANCER
#3120MOLECULAR GUIDE SYSTEM PEPTIDES AND USES THEREOF
#3121NUCLEIC ACID DELIVERY ENHANCER
#3122HUNTINGTIN (HTT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#3123ORAL DELIVERY OF OLIGONUCLEOTIDES
#3124DISRUPTING GENOMIC COMPLEX ASSEMBLY IN FUSION GENES
#3125Adeno-Associated Viral Vectors for Crossing the Human Blood Brain Barrier
#3126FLUID DELIVERY SYSTEMS AND METHODS OF TREATMENT
#3127Carbohydrate conjugate RNA agents and process for their preparation
#3128CONJUGATE OF GalNAc-OLIGONUCLEOTIDE FOR DELIVERY TO LIVER AND MANUFACTURING METHOD THEREOF
#3129Crispr enzymes and systems
#3130Temperature-based transient delivery of nucleic acids and proteins to cells and tissues
#3131VECTOR SYSTEM FOR EXPRESSING REGULATORY RNA
#3132Modified Guide RNAs for Gene Editing
#3133Modified antisense oligonucleotide for inhibition of FoxP3 expression
#3134PROMOTER HAVING HIGH ACTIVITY IN ACTIVATED T-CELL
#3135COMPOSITIONS AND METHODS FOR LOADING EXTRACELLULAR VESICLES WITH CHEMICAL AND BIOLOGICAL AGENTS/MOLECULES
#3136Oligonucleotide based ex vivo cell therapy
#3137STABILIZATION OF RNA FOR EXOGENOUS RNAi AGRICULTURAL APPLICATIONS AND FORMULATIONS
#3138Modified ribonucleic acids and uses thereof
#3139Dynamic pharmacokinetic-modifying anchors
#3140Inhibitors Of RNA Editing And Uses Thereof
#3141HYDROXYMETHYL-MODIFIED GAMMA-PNA COMPOSITIONS AND METHODS OF USE THEREOF
#3142ANTISENSE COMPOUNDS AND USES THEREOF
#3143MICRORNAS ENRICHED IN MEGAKARYOCYTIC EXTRACELLULAR VESICLES AND USES THEREOF
#3144Method and carrier complexes for delivering molecules to cells
#3145COMPOSITIONS CONTAINING NUCLEIC ACID NANOPARTICLES WITH MODULAR FUNCTIONALITY
#3146TREATMENT/PREVENTION OF DISEASE BY LINC COMPLEX INHIBITION
#3147THREE-DIMENSIONAL FLOW PATH STRUCTURE BODY AND NANOPARTICLE PRODUCTION METHOD USING SAME
#3148SYSTEMS AND METHODS FOR IN-VITRO MODELING OF NEURODEGENERATIVE DISEASES
#3149EPIGENETIC MODULATION OF GENOMIC TARGETS TO CONTROL EXPRESSION OF PWS-ASSOCIATED GENES
#3150TARGETING DELTAFOSB FOR TREATMENT OF DYSKINESIA
#3151METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#3152RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#3153EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#3154TREM COMPOSITIONS FOR CON-RARE CODONS AND RELATED USES
#3155COMPOSITIONS AND METHODS FOR REPROGRAMMING AGE-RESTRICTED NON-NEURONAL CELLS
#3156Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#3157METHOD OF STIMULATING PROLIFERATION OF A CELL
#3158COMPLEMENT COMPONENT C3 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3159PRODUCTS AND COMPOSITIONS
#3160ANTISENSE OLIGONUCLEOTIDE CAPABLE OF ALTERING SPLICING OF DUX4 pre-mRNA
#3161Antisense oligomers and methods of using the same for treating diseases associated with the acid alpha-glucosidase gene
#3162EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
#3163MicroRNA-33 inhibitors and use thereof in the treatment of pulmonary fibrosis
#3164Method for promoting differentiation of pluripotent stem cells by reducing undifferentiated state thereof
#3165MELANOPHILIN ANTISENSE OLIGONUCLEOTIDES
#31665`S-LNA nucleotides and oligonucleotides
#3167ANELLOVIRUS COMPOSITIONS AND METHODS OF USE
#3168INTRACELLULAR GENOMIC TRANSPLANT AND METHODS OF THERAPY
#3169ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA
#3170INSECT EXTRACELLULAR VESICLES FOR DELIVERY OF NUCLEIC ACIDS
#3171MAMMALIAN EXPRESSION VECTORS
#3172RAPID CHARACTERIZATION OF CAS ENDONUCLEASE SYSTEMS, PAM SEQUENCES AND GUIDE RNA ELEMENTS
#3173NUCLEIC ACID, COMPOSITION AND CONJUGATE COMPRISING THE SAME, PREPARATION METHOD AND USE THEREOF
#3174SIRNA FOR INHIBITING HTT GENE EXPRESSION, AND PRECURSOR AND APPLICATION THEREOF
#3175METHODS AND COMPOSITIONS FOR TYPE 2 DIABETES THERAPY
#3176CORRECTION OF EXON SKIPPING IN MONOCYTE-DERIVED CELLS FOR IMPROVED IMMUNE RESPONSE
#3177METHODS TO REPROGRAM SOMATIC CELLS TO ALTERNATIVE CELL FATES OR PRIMITIVE CELL STATES
#3178Molecular programming tools
#3179IMMOBILIZED POLY(N)POLYMERASE
#3180p63 inactivation for the treatment of heart failure
#3181LNCRNAS FOR THERAPY AND DIAGNOSIS OF CARDIAC HYPERTROPHY
#3182HYBRID NUCLEIC ACID MOLECULES AND THEIR USE
#3183OLIGONUCLEOTIDES FOR SYNGR-3 MODULATION
#3184LIPOSOMAL SPHERICAL NUCLEIC ACID (SNA) CONSTRUCTS FOR SPLICE MODULATION
#3185COMPOSITION FOR DIAGNOSIS OR TREATMENT OF A CONDITION ASSOCIATED WITH INCREASED ACTIVITY OF EIF4E COMPRISING AN EIF4E INHIBITOR
#3186GNAQ targeted dsRNA compositions and methods for inhibiting expression
#3187Oligonucleotide-ligand conjugates and process for their preparation
#3188MATERIALS AND METHODS FOR MODIFYING THE ACTIVITY OF T CELLS
#3189Exosome-Mediated Transfection for Delivery of Nucleic Acids
#3190RNAi insecticide materials and methods
#3191Method for the production of a catalytically active DNA molecule having improved activity and its use in a method of treating asthma
#3192TARGETING RLIM TO MODULATE BODY WEIGHT AND OBESITY
#3193Methods for treating SARS-CoV-2 infection
#3194METHODS FOR THE TREATMENT OF RETINAL DYSTROPHIES BY EXON-SKIPPING STRATEGY
#3195CHEMICALLY MODIFIED OLIGONUCLEOTIDES FOR RNA EDITING
#3196REDUCING BLOOD GLUCOSE, INSULIN RESISTANCE, OR HYPERLIPIDEMIA THROUGH RLIP76 PARTIAL DEPLETION
#3197USE OF REAGENT FOR DOWN-REGULATING CIRCULAR GENE EXPRESSION IN PREPARATION OF DRUGS FOR PREVENTING AND/OR TREATING PULMONARY FIBROSIS AND DRUG THEREOF
#3198METHODS OF TREATING OR SELECTING A TREATMENT FOR A SUBJECT RESISTANT TO TNF INHIBITOR USING A NLRP3 ANTAGONIST
#3199PARTICLES AND COMPOSITIONS COMPRISING THE SAME FOR TRANSFECTION
#3200SYSTEMS AND METHODS FOR GENERATING GENETIC INCOMPATIBILITY
#3201SYSTEMS AND METHODS FOR DETERMINING EFFECTS OF THERAPIES AND GENETIC VARIATION ON POLYADENYLATION SITE SELECTION
#3202MELANOGENESIS DETECTION METHOD USING FAM86A
#3203MODULATORY POLYNUCLEOTIDES
#3204A NUCLEIC ACID DELIVERY VECTOR COMPRISING A CIRCULAR SINGLE STRANDED POLYNUCLEOTIDE
#3205Antisense nucleic acid that induces skipping of exon 50
#3206ANTI-MIRNAS FOR THE TREATMENT OF LEIOMYOMA
#3207NUCLEIC ACID THAT INHIBITS EXPRESSION OF MEX3B GENE, MEX3B GENE EXPRESSION INHIBITING AGENT, METHOD FOR INHIBITING MEX3B GENE EXPRESSION, AND PROPHYLACTIC OR THERAPEUTIC AGENT FOR DISEASE CAUSED BY MEX3B GENE EXPRESSION
#3208Long Noncoding RNA Implicated in Cardiovascular Disease and Use Thereof
#3209COMBINATIONS OF SIRNAS WITH SIRNAS AGAINST SULF2 OR GPC3 FOR USE IN TREATING CANCER
#3210VASCULOGENIC FIBROBLASTS
#3211COMPOSITIONS AND METHODS FOR IN VIVO GENE EDITING
#3212OLIGONUCLEOTIDES AND METHODS OF USE FOR TREATING NEUROLOGICAL DISEASES
#3213TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#3214Polynucleotide encoding modified CAS9 protein
#3215CD71 binding fibronectin type III domains
#3216Modified RNAi agents
#3217Tumor-Targeting Polypeptide Nanoparticle Delivery System for Nucleic Acid Therapeutics
#3218FACTOR IX GENE THERAPY
#3219METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS
#3220NOVEL EUKARYOTIC CELLS AND METHODS FOR RECOMBINANTLY EXPRESSING A PRODUCT OF INTEREST
#3221Methods and systems for guide RNA design and use
#3222PROMOTERS FROM CORYNEBACTERIUM GLUTAMICUM
#3223OLIGONUCLEOTIDE, AND TARGET RNA SITE-SPECIFIC EDITING METHOD
#3224ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATING PENDRED SYNDROME
#3225PLATFORM FOR THE INDUCTION & MAINTENANCE OF GROUND STATE PLURIPOTENCY
#3226Methods of delivering an oligonucleotide to a subject having facioscapulohumeral muscular dystrophy
#3227NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#3228Modified peptide nucleic acid compositions
#3229Methicillin-Resistant Staphylococcus Aureus Mutant Strain And Use Thereof
#3230Pharmaceutical composition for treatment and prevention of chronic disease
#3231SYNTHETIC LIPID-LIKE MATERIALS FOR BRAIN DELIVERY
#3232DNAZYMES FOR DETECTING LEGIONELLA PNEUMOPHILA
#3233Methods for genetic control of insect infestations in plants and compositions thereof
#3234Extended dicer substrate agents and methods for the specific inhibition of gene expression
#3235LNCRNAS FOR THERAPY AND DIAGNOSIS OF CARDIAC HYPERTROPHY
#3236COMPOUNDS AND METHODS FOR REDUCING SNCA EXPRESSION
#3237Methods and Compositions for Selecting siRNA of Improved Functionality
#3238Gene-regulating compositions and methods for improved immunotherapy
#3239IMPROVED ANTIBODY-OLIGONUCLEOTIDE CONJUGATE
#3240Nucleic acid-polypeptide compositions and methods of inducing exon skipping
#3241SEQUENCE-SPECIFIC IN VIVO CELL TARGETING
#3242A PHARMACEUTICAL COMPOSITION OF S1PR MODULATORS
#3243ASSAYS AND METHODS FOR DETERMINING ACTIVITY OF A THERAPEUTIC AGENT IN A SUBJECT
#3244REGULATABLE EXPRESSION SYSTEMS
#3245COMPOSITIONS AND METHODS FOR MITIGATION OF ISCHEMIC REPERFUSION INJURY
#3246RNA-Editing Enzyme-Recruiting Oligonucleotides and Uses Thereof
#3247UNIFIED PORTAL FOR REGULATORY AND SPLICING ELEMENTS FOR GENOME ANALYSIS
#3248PROCESS OF DELIVERING SMALL RNAS TO SPERM
#3249DELIVERY OF OLIGONUCLEOTIDES TO THE STRIATUM
#3250ANTISENSE RNA EDITING OLIGONUCLEOTIDES COMPRISING CYTIDINE ANALOGS
#3251RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF
#3252A NEUROPILIN ANTAGONIST IN COMBINATION WITH A P38ALPHA-KINASE INHIBITOR FOR THE TREATMENT OF CANCER
#3253METHODS AND COMPOSITIONS FOR EDITING RNAS
#3254DOUBLE-STRANDED NUCLEIC ACID COMPLEX AND USE THEREOF
#3255Compositions, methods, modules and instruments for automated nucleic acid-guided nuclease editing in mammalian cells via viral delivery
#3256EVOLVED CAS9 VARIANTS AND USES THEREOF
#3257METHODS OF TREATING CANCER BY TARGETING ZSCAN4 ACTIVITY IN CANCER STEM CELLS
#3258Oligonucleotide compositions and methods of making the same
#3259OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#3260SKELETAL MYOBLAST PROGENITOR CELL LINEAGE SPECIFICATION BY CRISPR/CAS9-BASED TRANSCRIPTIONAL ACTIVATORS
#3261SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3262METHODS AND COMPOSITIONS FOR MICROBIAL DELIVERY OF DOUBLE STRANDED RNA
#3263MULTI-INPUT MIRNA SENSING WITH CONSTITUTIVE ERNS TO REGULATE MULTI-OUTPUT GENE EXPRESSION IN MAMMALIAN CELLS
#3264GALNAC CLUSTER PHOSPHORAMIDITE AND TARGETED THERAPEUTIC NUCLEOSIDES
#3265COMPOSITIONS AND METHODS FOR RNA INTERFERENCE
#3266Novel Retinitis Pigmentosa Treatment
#3267NOVEL EUKARYOTIC CELLS AND METHODS FOR RECOMBINANTLY EXPRESSING A PRODUCT OF INTEREST
#3268COMPOUNDS AND METHODS FOR MODULATING ANGIOTENSINOGEN EXPRESSION
#3269DIAGNOSTIC AND THERAPEUTIC USES OF COMPOSITIONS COMPRISING PURIFIED, ENRICHED POTENT EXOSOMES CONTAINING DISEASE-BASED AND THERAPY BASED SIGNATURE CARGO
#3270METHODS FOR TREATING MUSCULAR DYSTROPHY
#3271METHODS FOR TREATING MUSCULAR DYSTROPHY USING INHIBITORY OLIGONUCLEOTIDES TO CD49D
#3272HUMAN HEAD AND NECK CANCER TREATMENT
#3273NUCLEIC ACID-CONTAINING LIPID PARTICLES AND RELATED METHODS
#3274RNA-based control of powdery mildew
#3275Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro
#3276Defined multi-conjugates oligonucleotides
#3277Compounds and methods for modulating ATXN1
#3278Modified RNA agents with reduced off-target effect
#3279Nucleic acids for inhibiting expression of LPA in a cell
#3280Products and compositions
#3281COMPOSITIONS AND METHODS FOR MODULATING SPLICING AND PROTEIN EXPRESSION
#3282ANTISENSE OLIGONUCLEOTIDE THERAPY FOR CANCER
#3283TRANS-CYCLOOCTENE LABELED ANTISENSE OLIGONUCLEOTIDES, RADIO LABELED TETRAZINE AND METHODS
#3284METHODS AND COMPOSITIONS FOR GENE SPECIFIC DEMETHYLATION AND ACTIVATION
#3285Methods to detect motor neuron disease comprising micro-RNAs
#3286COMPOUNDS AND METHODS FOR REDUCING SPDEF EXPRESSION
#3287MATERIALS AND METHODS FOR TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS
#3288CANCER TREATMENT THROUGH RLIP76 PARTIAL DEPLETION
#3289EFFICIENT METHOD FOR PREPARING PPR PROTEIN AND USE OF THE SAME
#3290Tetragalnac and peptide containing conjugates and methods for delivery of oligonucleotides
#3291Use of Thermostable RNA Polymerases to Produce RNAs Having Reduced Immunogenicity
#3292RNA-BASED THERAPEUTIC METHODS TO PROTECT ANIMALS AGAINST PATHOGENIC BACTERIA AND / OR PROMOTE BENEFICIAL EFFECTS OF SYMBIOTIC AND COMMENSAL BACTERIA
#3293METHODS OF CANCER TREATMENT BY DELIVERY OF siRNAs AGAINST BCLXL AND MCL1 USING A POLYPEPTIDE NANOPARTICLE
#3294Muscle targeting complexes and uses thereof for treating dystrophinopathies
#3295GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#3296MULTILAMELLAR RNA NANOPARTICLES
#3297High performance multi-input microRNA sensors and uses thereof
#3298NOVEL CRISPR DNA TARGETING ENZYMES AND SYSTEMS
#3299METHODS OF INDUCING INSULIN PRODUCTION
#3300P38 KINASE INHIBITORS REDUCE DUX4 AND DOWNSTREAM GENE EXPRESSION FOR THE TREATMENT OF FSHD