109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
Treatment of liver diseases with cell death inducing DFFA like effector B (CIDEB) inhibitors
#3302Compositions and Methods for MYC Messenger RNA Inhibitors
#3303COMPOSITIONS AND METHODS FOR DETECTING AND TREATING INSULIN RESISTANCE
#3304LONG NON-CODING RNA IN CANCER
#3305COMPOUNDS AND METHODS USEFUL FOR MODULATING GENE SPLICING
#3306MOLECULAR TARGETED NUCLEIC ACID MEDICINE FOR GASTRIC CANCER
#3307EXON 44-TARGETED NUCLEIC ACIDS AND RECOMBINANT ADENO-ASSOCIATED VIRUS COMPRISING SAID NUCLEIC ACIDS FOR TREATMENT OF DYSTROPHIN-BASED MYOPATHIES
#3308OLIGONUCLEOTIDE THERAPY FOR STARGARDT DISEASE
#3309COMPOSITIONS AND METHODS OF NUCLEIC ACID-TARGETING NUCLEIC ACIDS
#3310METHOD FOR PRODUCING PARVALBUMIN-POSITIVE NERVE CELLS, CELL, AND DIFFERENTIATION INDUCER
#3311VH4 antibodies and compositions comprising the same
#3312COMPOSITIONS AND METHODS FOR TREATING SICKLE CELL DISEASE
#3313COMBINATION THERAPY FOR SPINAL MUSCULAR ATROPHY
#3314Exon skipping oligomer conjugates for muscular dystrophy
#3315CHIMERIC MOLECULE, PHARMACEUTICAL COMPOSITION, METHOD FOR CLEAVING TARGET NUCLEIC ACID, AND KIT FOR TARGET NUCLEIC ACID CLEAVAGE OR DIAGNOSIS
#3316METHOD AND COMPOSITION FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#3317PRODUCTION OF VANILLIN-GLUCOSIDE FROM LIGNIN-DERIVED CARBON
#3318METHOD FOR ENCODING DNA/RNA SEQUENCES BASED ON BIDIRECTIONAL TRINUCLEOTIDE POSITION-SPECIFIC PROPENSITIES AND POINTWISE JOINT MUTUAL INFORMATION
#3319METHODS AND COMPOSITIONS FOR TREATING MALIGNANT TUMORS ASSOCIATED WITH KRAS MUTATION
#3320NEW TREATMENTS INVOLVING MIRNA-193A
#3321COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#3322RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING CHEMICALLY MODIFIED SHORT INTERFERING NUCLEIC ACID (SINA)
#3323COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#3324ß-AMYLOID CYCLIC RIBONUCLEIC ACID, POLYPEPTIDE, AND APPLICATION THEREOF
#3325ENHANCED TRANSDUCTION OF AAV VECTORS ENCODING MICRORNAS
#3326Altering microbial populations and modifying microbiota
#3327COMPOSITIONS AND METHODS FOR DECREASING INTRAOCULAR PRESSURE
#3328Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#3329Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#3330Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#3331COMPOSITIONS AND METHODS TO CONTROL INSECT PESTS
#3332Creation of herbicide resistant gene and use thereof
#3333NUCLEIC ACID CONSTRUCT COMPRISING 5' UTR STEM-LOOP FOR IN VITRO AND IN VIVO GENE EXPRESSION
#3334COMPOSITIONS AND METHODS OF USING C/EBP ALPHA SARNA
#3335MEDICAL USES, METHODS AND USES
#3336Recombinant virus products and methods for inducing DUX4 exon skipping
#3337METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#3338RNA INTERFERENCE-INDUCING NUCLEIC ACID INHIBITING NONCANONICAL TARGETS OF MICRO RNA, AND USE FOR SAME
#3339TREATMENT OF GENETIC DISORDERS ASSOCIATED WITH DNA REPEAT INSTABILITY
#3340HSD17B13 variants and uses thereof
#3341Method for purifying an enveloped virus
#3342Gene-regulating compositions and methods for improved immunotherapy
#3343BIODEGRADABLE CATIONIC POLYMERS AND USES THEREOF
#3344SPLICE MODULATING OLIGONUCLEOTIDES TARGETING RECEPTOR FOR ADVANCED GLYCATION END PRODUCTS AND METHODS OF USE
#3345COMPOSITIONS AND METHODS FOR THE TREATMENT OF LEUKODYSTROPHY AND WHOLE ANIMAL AND CELLULAR MODELS FOR IDENTIFYING EFFICACIOUS AGENTS FOR TREATMENT OF THE SAME
#3346Micro-RNAs and compositions comprising same for the treatment and diagnosis of serotonin-, adrenalin-, noradrenalin-, glutamate-, and corticotropin-releasing hormone- associated medical conditions
#3347Methods to determine the effect of an agent on mammalian embryonic development
#3348SENSOR AND SENSING SYSTEM
#3349Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#3350METHODS AND COMPOSITIONS FOR MODIFYING CYTOKININ OXIDASE LEVELS IN PLANTS
#3351INCREASING ATOH1 LIFE TO DRIVE SENSORINEURAL HAIR CELL DIFFERENTIANTION
#3352COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#3353OLIGONUCLEOTIDE ANTAGONISTS FOR RNA GUIDED GENOME EDITING
#3354Inhibitors of microRNA 451a for Treatment of Endometriosis
#3355FUNCTIONAL NUCLEIC ACID MOLECULES UPREGULATING THE TRANSLATION OF A FRATAXIN MRNA
#3356VECTORS AND COMPOSITIONS FOR TREATING HEMOGLOBINOPATHIES
#3357CONTROL OF MAMMALIAN GENE DOSAGE USING CRISPR
#3358EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#3359Anti-inflammatory treatment via inhibition of endothelial cell kinesin light chain 1, variant 1 (KLC1C)
#3360REVERSIR™ compounds
#3361MATERIALS AND METHODS FOR TREATMENT OF HEMOGLOBINOPATHIES
#3362RECOMBINANT AD35 VECTORS AND RELATED GENE THERAPY IMPROVEMENTS
#3363MICELLAR NANOPARTICLES AND USES THEREOF
#3364COMBINATION THERAPY FOR THE TREATMENT OF AUTOIMMUNE DISEASES
#3365Small peptide compositions and uses thereof
#3366ANTI-INFECTION EFFECTS OF HNRNPA2B1 AND USE THEREOF
#3367REDUCTION OF BONE RESORPTION, ESPECIALLY IN CHRONIC JOINT DISEASES
#3368Methods of Treating Transthyretin (TTR) Mediated Amyloidosis
#3369MUTANT CALRETICULIN FOR THE DIAGNOSIS OF MYELOID MALIGNANCIES
#3370Genetic elements driving circular RNA translation and methods of use
#3371METHODS FOR PRODUCING CELL POPULATIONS WITH INCREASED NUCLEIC ACID UPTAKE
#3372ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#3373Compositions and methods for disrupting the molecular mechanisms associated with mitochondrial dysfunction and neurodegenerative disease
#3374METHOD FOR REDUCING TOXICITY OF ANTISENSE NUCLEIC ACIDS
#3375Enhanced oligonucleotides for inhibiting RTEL1 expression
#3376O-methyl rich fully stabilized oligonucleotides
#3377OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA
#3378Methods and compositions for inhibiting PMP22 expression
#3379Regenerative Therapy Based on miRNA-302 Mimics for Enhancing Host Recovery from Pneumonia Caused by Streptococcus pneumoniae
#3380EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
#3381Inhibition of nucleic acid polymerases by endonuclease V-cleavable circular oligonucleotide ligands
#3382Inhibition of DNA polymerases by uracil-DNA glycosylase-cleavable oligonucleotide ligands
#3383METHODS AND COMPOSITIONS RELATING TO ANTI-NUCLEOLIN RECOMBINANT IMMUNOAGENTS
#3384Agents and Methods for Treating Viral Infections
#3385GENE THERAPY FOR RETINAL DISEASE
#3386AAV DELIVERY OF NUCLEOBASE EDITORS
#3387PEGylated synthetic KL4 peptide, Compositions and Methods Thereof
#3388TRANSFECTION METHOD
#3389IMMUNOTHERAPEUTIC CONSTRUCTS AND METHODS OF THEIR USE
#3390SEX-LINKED RNAI INSECTICIDE MATERIALS AND METHODS
#3391Adeno-Associated Virus Virions with Variant Capsid and Methods of Use Thereof
#3392Compositions and Methods for Monitoring, Diagnosis, Detection and Treatment of Cancer
#3393ANALYSIS OF NUCLEIC ACIDS ASSOCIATED WITH SINGLE CELLS USING NUCLEIC ACID BARCODE
#3394Modulators of MALAT1 expression
#3395TREATMENT OF HEART FAILURE IN HUMAN SUBJECTS
#3396COMPOUNDS AND METHODS FOR REDUCING FUS EXPRESSION
#3397NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#3398ENGINEERED ITR SEQUENCES AND METHODS OF USE
#3399COMPOSITIONS AND METHODS FOR MODULATING TAU EXPRESSION
#3400Lipid formulated compositions and methods for inhibiting expression of serum amyloid a gene
#3401TARGETED RNA EDITING BY LEVERAGING ENDOGENOUS ADAR USING ENGINEERED RNAS
#3402FUSION PROTEIN FOR NATURAL KILLER CELL SPECIFIC CRISPR/CAS SYSTEM AND USE THEREOF
#3403OPTIMIZED GENETIC TOOL FOR MODIFYING BACTERIA
#3404Targeted replacement of endogenous T cell receptors
#3405Altering microbial populations and modifying microbiota
#3406RNA targeting methods and compositions
#3407CRISPR GUIDE SELECTION
#3408Compositions and methods for monitoring, diagnosis, prognosis, detection, and treatment of cancer
#3409Use of novel miRNA-binding site cassettes for antigen-presenting cell detargeting of transgene expression by rAAV gene therapy vectors
#3410Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#3411Antisense oligonucleotides for the treatment of Leber congenital amaurosis
#3412NUCLEIC ACID COMPOSITIONS AND METHODS OF MULTI-EXON SKIPPING
#3413PROTECTIVE ELEMENTS FOR NUCLEIC ACID SYNTHETIC BIOLOGY
#3414MINIGENE THERAPY
#3415NUCLEIC ACID CARRIER AND METHOD FOR ADMINISTERING NUCLEIC ACID
#3416NANOGOLD-DNA BIOCONJUGATES AND METHODS OF USE THEREOF
#3417ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA
#3418METHODS AND COMPOSITIONS FOR TREATING PULMONARY ARTERIAL HYPTERNSION
#3419Compositions and methods for organ specific delivery of nucleic acids
#3420USE OF CD9 AS A BIOMARKER AND AS A BIOTARGET IN GLOMERULONEPHRITIS OR GLOMERULOSCLEROSIS
#3421SINGLE INPUT MULTIPLEX DECISION SYSTEMS AND METHODS OF USING THE SAME
#3422Methods for production of strictosidine aglycone and monoterpenoid indole alkaloids
#3423Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA
#3424EUKARYOTIC SEMI-SYNTHETIC ORGANISMS
#3425USES OF TREM COMPOSITIONS TO MODULATE TRNA POOLS
#3426MICRO-RNA SITE BLOCKING OLIGONUCLEOTIDES FOR THE TREATMENT OF EPILEPTIC ENCEPHALOPATHY AND NEURODEVELOPMENTAL DISORDERS
#3427A Ribozyme Comprising a Target-Binding Domain
#3428SERPIN FAMILY F MEMBER 2 (SERPINF2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3429MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#3430COMPOSITIONS AND METHODS FOR EDITING BETA-GLOBIN FOR TREATMENT OF HEMAGLOBINOPATHIES
#3431OLIGONUCLEOTIDES FOR DGAT2 MODULATION
#3432COMPOUND, METHOD AND PHARMACEUTICAL COMPOSITION FOR MODULATING EXPRESSION OF DUX4
#3433DNA-CUTTING AGENT BASED ON CAS9 PROTEIN FROM THE BACTERIUM PASTEURELLA PNEUMOTROPICA
#3434CLEAVING PRE-FUSION STATE SARS-COV-2 SPIKE PROTEIN
#3435Gene LBA5 for regulating lateral shoot angles, growth habits, and plant architecture of L., and use thereof
#3436Methods for efficient delivery of therapeutic molecules in vitro and in vivo
#3437Coordinating gene expression using RNA destabilizing elements
#3438THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#3439Compositions and methods for the delivery of nucleic acids
#3440Compositions and Methods for Modulating MECP2 Expression
#3441METHODS AND COMPOSITIONS FOR TREATING MELANOMA
#3442Methods for production and quantification of unique molecular identifier-labeled beads
#3443Cell-specific expression of modRNA
#3444SYNTHETIC PRODUCTION OF SINGLE-STRANDED ADENO ASSOCIATED VIRAL DNA VECTORS
#3445NUCLEIC ACID DRUG SUPPRESSING PRODUCTION OF MYOSTATIN GENE MRNA
#3446METHODS OF TREATING DISEASES ASSOCIATED WITH CELLS EXHIBITING ER STRESS OR WITH NEURAL TISSUE DAMAGE
#3447MEDIATORS OF GENE SILENCING
#3448METHOD FOR CONTROLLING MICRORNA EXPRESSION
#3449Treatment of liver diseases with cell death inducing DFFA like effector B (CIDEB) inhibitors
#3450Gene-regulating compositions and methods for improved immunotherapy
#3451NUCLEIC ACID CONJUGATES AND USES THEREOF
#3452Sequence specific antimicrobials
#3453Sequence specific antimicrobials
#3454Sequence specific antimicrobials
#3455NEW THERAPY
#3456Therapeutic pharmaceutical composition for cancer including miRNA
#3457IONIZABLE CATIONIC LIPIDS AND LIPID NANOPARTICLES, AND METHODS OF SYNTHESIS AND USE THEREOF
#3458VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF PF-ILD AND IPF
#3459METHOD OF PRODUCING MICROBIAL OIL CONTAINING FATTY ACIDS OBTAINED FROM STRAMENOPILE
#3460METHODS FOR TREATMENT OF POLYCYSTIC KIDNEY DISEASE
#3461TARGETING MISSPLICED TRANSCRIPTS IN GENETIC DISORDERS
#3462Targeted inhibition using engineered oligonucleotides
#3463Targeted inhibition using engineered oligonucleotides
#3464RESTORATION OF THE CFTR FUNCTION BY SPLICING MODULATION
#3465ANTISENSE OLIGONUCLEOTIDES FOR THE TREATMENT OF USHER SYNDROME
#3466Therapeutic Targeting of a microRNA to Treat Duchenne Muscular Dystrophy
#3467Oral delivery of antisense conjugates targeting PCSK9
#3468DUAL TARGETING siRNA AGENTS
#3469MODULATION OF TRANSTHYRETIN EXPRESSION
#3470COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#3471MODULATION OF APOLIPOPROTEIN C-III (APOCIII) EXPRESSION IN LIPOPROTEIN LIPASE DEFICIENT (LPLD) POPULATIONS
#3472METHODS AND COMPOSITIONS FOR BARCODING NUCLEIC ACID LIBRARIES AND CELL POPULATIONS
#3473Variant CAS12 proteins with improved DNA cleavage selectivity and methods of use
#3474Thermostable CAS9 nucleases
#3475MATERIALS AND METHODS FOR TREATMENT OF HEMOGLOBINOPATHIES
#3476Treatment of primary ciliary dyskinesia with synthetic messenger RNA
#3477GENE THERAPIES FOR LYSOSOMAL DISORDERS
#3478Treatment of amyotrophic lateral sclerosis (ALS)
#3479ORAL DELIVERY OF OLIGONUCLEOTIDES
#3480SIRT1-SARNA COMPOSITIONS AND METHODS OF USE
#3481Nanoparticle to target cancer
#3482IMAGING-BASED POOLED CRISPR SCREENING
#3483SYSTEM FOR GENOME EDITING
#3484RAAV-based compositions and methods
#3485Antisense oligonucleotide for targeting progranulin
#3486Antisense oligonucleotides for the treatment of Stargardt disease
#3487Compositions and Methods for Inhibiting Cancers and Viruses
#3488Genetically-modified immune cells comprising a microRNA-adapted shRNA (shRNAmiR)
#3489LIPIDS AND LIPID NANOPARTICLE FORMULATIONS FOR DELIVERY OF NUCLEIC ACIDS
#3490COMPOSITIONS USEFUL IN TREATMENT OF RETT SYNDROME
#3491Agent for use in the treatment of glioma
#3492Compositions and methods for organ-protective expression and modulation of coding ribonucleic acids
#3493Therapeutic pharmaceutical composition for cancer including miRNA
#3494HIGH DENSITY LIPOPROTEIN BINDING PROTEIN (HDLBP/VIGILIN) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#3495MOLECULAR MARKER DETECTION AND REGULATING METHODS IN DE-SERVITIZATION STATE OF CELLS
#3496Crispr enzymes and systems
#3497RETROVIRAL VECTOR HAVING IMMUNE-STIMULATING ACTIVITY
#3498Curing for recursive nucleic acid-guided cell editing
#3499TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#3500TAU-TARGETING OLIGONUCLEOTIDE GAPMERS
#3501NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL
#3502Antisense oligonucleotide and double stranded RNAS for control of hemipteran and lepidopteran pests
#3503Oversubscription scheduling
#3504RNA interference mediated inhibition of gene expression using short interfering nucleic acids (siNA)
#3505Methods for preventing and treating or diagnosing coronavirus infection
#3506COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION
#3507Compositions for modulating Ataxin 2 expression
#3508OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#3509OLIGONUCLEOTIDES AND METHODS FOR THE TREATMENT OF AGE-RELATED MACULAR DEGENERATION
#3510SIMULTANEOUS MULTIPLEX GENOME EDITING IN YEAST
#3511Novel Process for Preparing Rhenium Chelated MAG3 Oligonucleotides
#3512Compositions and methods for the treatment of cancer using a CD8 engineered T cell therapy
#3513HEMOPHILIA B RAT MODEL
#3514Inbred watermelon line WDL0090
#3515IMPROVEMENTS RELATING TO CELL TRANSFECTION
#3516AAV-CAS13D VECTORS AND USES THEREOF
#3517Diplospory gene
#3518Linkage modified oligomeric compounds and uses thereof
#3519NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND CONJUGATE, PREPARATION METHOD AND USE
#3520Use of miR-18b for prevention, treatment, or diagnosis of muscle disease and neuromuscular disease
#3521MODIFYING THE SPECIFICITY OF NON-CODING RNA MOLECULES FOR SILENCING GENES IN EUKARYOTIC CELLS
#3522METHODS AND COMPOSITIONS FOR CORRECTED ABERRANT SPLICE SITES
#3523OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#3524Compositions and Methods for Treatment of Disorders Associated with Repetitive DNA
#3525NOVEL Cas ENZYME AND SYSTEM, AND USE THEREOF
#3526INTRACELLULAR TARGETING OF MOLECULES
#3527Correction of Beta-Thalassemia Phenotype by Genetically Engineered Hematopoietic Stem Cell
#3528COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#3529RIBOSOME VARIANTS FOR SEQUENCE DEFINED POLYMER SYNTHESIS
#3530Methods for increasing observed editing in bacteria
#3531Treatment and diagnosis of inflammatory disorders
#3532MicroRNA-198 as a tumor suppressor in ovarian cancer
#3533ENDOSOMAL CLEAVABLE LINKERS
#3534Oligonucleotides for modulating Tau expression
#3535Antisense Oligonucleotides Targeting ATXN3
#3536CALCINEURIN INHIBITOR RESISTANT IMMUNE CELLS FOR USE IN ADOPTIVE CELL TRANSFER THERAPY
#3537DOUBLE-STRANDED NUCLEIC ACID INHIBITOR MOLECULES WITH SHORTENED SENSE STRANDS
#3538CRISPR/CAS9 GENE EDITING OF ATXN2 FOR THE TREATMENT OF SPINOCEREBELLAR ATAXIA TYPE 2
#3539Multicistronic miRNA delivery for cardiac reprogramming
#3540AIM2 INHIBITORS AND USES THEREOF
#3541POLYMER NANOPARTICLE AND DNA NANOSTRUCTURE COMPOSITIONS AND METHODS FOR NON-VIRAL DELIVERY
#3542COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING VIRAL INFECTIONS
#3543Compositions comprising riboregulators and methods of use thereof
#3544ADENOSINE DEAMINASE BASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE IN A TARGET SEQUENCE
#3545Modulation of prekallikrein (PKK) expression
#3546Antisense oligonucleic acid
#3547NANOSYSTEM BASED ON MICRORNA FOR TREATING OBSESITY
#3548CONTROL OF INSECT PESTS USING RNA MOLECULES
#3549IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#3550Nucleic acids for inhibiting expression of LPA in a cell
#3551Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use
#3552MicroRNA expression promoting agent and food or beverage for promoting expression of microRNA
#3553Method for constructing functional exosomes capable of efficiently loading specific miRNA
#3554Methods of intravenouisly delivering anti-transferrin antibody/oligonucleotide complexes to subjects having muscular dystrophy
#3555Nucleic acid compound and oligonucleotide
#3556BLOCK COPOLYMERS AND USES THEREOF
#3557PLAKOPHILIN-2 (PKP2) GENE THERAPY USING AAV VECTOR
#3558Plakophilin-2 (PKP2) gene therapy using AAV vector
#3559Ventricular arrhythmias and related methods
#3560NOVEL METHOD FOR MONITORING ENDOMETRIOSIS AND ASSOCIATED DISORDERS
#3561Nucleic acid-guided nucleases
#3562Methods for reducing Ataxin-2 expression
#3563RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#3564ANGPTL4 oligonucleotides influencing the regulation of the fatty acid metabolism
#3565SYNTHETIC TRANSFER RNA WITH EXTENDED ANTICODON LOOP
#3566INHIBITOR OF MIR-129 AND USES THEREOF
#3567NOVEL RNA TRANSCRIPT
#3568Modulatory polynucleotides
#3569Extended dicer substrate agents and methods for the specific inhibition of gene expression
#3570NUCLEIC ACID COMPLEX FOR MODULATING IHH EXPRESSION
#3571NRL EXPRESSION REDUCING OLIGONUCLEOTIDES, COMPOSITIONS CONTAINING THE SAME, AND METHODS OF THEIR USE
#3572ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#3573ANTISENSE NUCLEIC ACIDS
#3574COMPOSITIONS COMPRISING ALTERNATING 2'-MODIFIED NUCLEOSIDES FOR USE IN GENE MODULATION
#3575POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF
#3576HIGH THROUGHPUT GENE EDITING SYSTEM AND METHOD
#3577Compositions for the Multiplexed Detection of Viruses
#3578OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#3579RNA STABILIZATION
#3580CPF1 COMPLEXES WITH REDUCED INDEL ACTIVITY
#3581AN OPTIMIZED ACCEPTOR SPLICE SITE MODULE FOR BIOLOGICAL AND BIOTECHNOLOGICAL APPLICATIONS
#3582Method for stimulating axonal regeneration
#3583NEOANTIGEN ENGINEERING USING SPLICE MODULATING COMPOUNDS
#3584BIFUNCTIONAL VECTORS ALLOWING BCL11A SILENCING AND EXPRESSION OF AN ANTI-SICKLING HBB AND USES THEREOF FOR GENE THERAPY OF B-HEMOGLOBINOPATHIES
#3585SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
#3586PROCESS CONTROL IN CELL BASED ASSAYS
#3587Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#3588SYSTEM AND METHOD FOR LIGHT-REGULATED OLIGOMERIZATION AND PHASE SEPARATION OF FOLDED DOMAINS AND RNA GRANULE-ASSOCIATED PROTEIN DOMAINS FOR DRUG- BASED SCREENING APPLICATIONS
#3589NOVEL NUCLEIC ACID MOLECULES AND THEIR USE IN THERAPY
#3590HETERO DOUBLE-STRANDED antimiR
#3591INCREASING GENOME STABILITY AND REPROGRAMMING EFFICIENCY OF INDUCED PLURIPOTENT STEM CELLS
#3592CHMP2A as a Regulator of Natural Killer Cell-Mediated Activity
#3593ANTISENSE OLIGONUCLEOTIDE-BASED PROGRANULIN AUGMENTATION THERAPY IN NEURODEGENERATIVE DISEASES
#3594FATTY ACID SYNTHASE, INHIBITORS AND MODIFICATIONS THEREOF AND ITS USE
#3595Compounds and methods for modulating angiotensinogen expression
#3596Compositions and methods for targeted RNA delivery
#3597MUC1 PARALLEL CAR (pCAR) THERAPEUTIC AGENTS
#3598Particle-mediated delivery of biologics
#3599Therapeutic targets for facioscapulohumeral muscular dystrophy
#3600Oligonucleotides for inducing paternal UBE3A expression