109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTION
#4202Application of microRNA-210 inhibitor in preparation of drugs for treating inflammatory skin diseases
#4203Compositions for Transfecting Resistant Cell Types
#4204COMPOSITIONS AND METHODS FOR THE TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#4205Methods and products for genetic engineering
#4206ANTISENSE NUCLEIC ACIDS
#4207Engineered Exosomes for Medical Applications
#4208METHODS AND COMPOUNDS FOR TREATMENT OF LYMPHOCYTE-RELATED DISEASES AND CONDITIONS
#4209ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA
#4210USE OF MYOSTATIN INHIBITORS AND COMBINATION THERAPIES
#4211Methods for treating hepatitis B infection
#4212COMPOSITIONS AND METHODS FOR THE TREATMENT OF ACUTE AND CHRONIC PRURITIS
#4213METHOD FOR TREATING NEURODEGENERATIVE DISEASES
#4214Homologous Recombination Reporter Construct and Uses Thereof
#4215AAV VARIANTS WITH ENHANCED TROPISM
#4216Targeting microRNA-101-3p in cancer therapy
#4217Small cell lung cancer therapeutic agent containing oligonucleotide
#4218Compounds and methods for modulating UBE3A-ATS
#4219Methods and compositions for sensitization of tumor cells to immune therapy
#4220Methods and compositions for modulating lncRNAs and methods of treatment based on lncRNA expression
#4221Short hairpin RNA compositions, methods of making and applications thereof
#4222Methods and Compositions for the Single Tube Preparation of Sequencing Libraries Using Cas9
#4223Compositions and methods for evading bacterial defense mechanisms
#4224ENGINEERING OF SYSTEMS, METHODS AND OPTIMIZED GUIDE COMPOSITIONS WITH NEW ARCHITECTURES FOR SEQUENCE MANIPULATION
#4225COMPOSITIONS AND METHODS OF USE OF CRISPR-CAS SYSTEMS IN NUCLEOTIDE REPEAT DISORDERS
#4226FIBER ASSEMBLY AND USE THEREOF
#4227KIDNEY DISEASE TARGETS AND USES THEREOF
#4228Compound usable as cationic lipid
#4229Therapeutic bacterial composition
#4230Methods for diagnosis and treatment of type 1 diabetes
#4231COMPOSITIONS FOR CONFERRING TOLERANCE TO VIRAL DISEASE IN SOCIAL INSECTS, AND THE USE THEREOF
#4232Nucleic acid, pharmaceutical composition and conjugate containing nucleic acid, and use thereof
#4233MICRORNA-134 BIOMARKER
#4234CRISPR EFFECTOR SYSTEM BASED AMPLIFICATION METHODS, SYSTEMS, AND DIAGNOSTICS
#4235OLIGONUCLEOTIDE-BASED PROTEOLYSIS TARGETING CHIMERA
#4236Methods of Managing Nucleic Acid Replication, Expression, and Cleavage Using CRISPR Associated Nucleases
#4237RNA MOLECULES COMPRISING NON-CANONICAL BASE PAIRS
#4238SYNTHETIC GUIDE MOLECULES, COMPOSITIONS AND METHODS RELATING THERETO
#4239MODIFICATION OF SMALL RNAS FOR THERAPEUTIC USES
#4240METHODS AND COMPOSITIONS FOR TARGETING PD-L1
#4241Serpina1 iRNA compositions and methods of use thereof
#4242Virus-like particles and use thereof
#4243Compounds and methods for the modulation of proteins
#4244Sideroflexins as mitochondrial serine transporters
#4245Lipid formulations for nucleic acid delivery
#4246Artificial exosome composition and related methods
#4247Compositions and methods for mitigating pest infestation with
#4248RNA INTERFERENCE IN DERMAL AND FIBROTIC INDICATIONS
#4249Compositions and methods of inhibiting gene expression in a lung
#4250COMPOSITION COMPRISING ANTISENSE OLIGONUCLEOTIDE AND USE THEREOF FOR TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY
#4251CORRECTION OF DYSTROPHIN EXON 43, EXON 45, OR EXON 52 DELETIONS IN DUCHENNE MUSCULAR DYSTROPHY
#4252ANTISENSE OLIGONUCLEOTIDES TARGETING TIA1
#4253METHOD OF USING CUT&RUN OR CUT&TAG TO VALIDATE CRISPR-CAS TARGETING
#4254Complement component C3 iRNA compositions and methods of use thereof
#4255Modified compounds and uses thereof
#4256MUSCLE-TARGETING COMPLEXES AND USES THEREOF
#4257AAV CARDIAC GENE THERAPY FOR CARDIOMYOPATHY
#4258ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#4259CHIMERIC PEPTIDES FOR ANTISENSE DELIVER
#4260COMPOSITIONS AND METHODS FOR INHIBITION OF LINEAGE SPECIFIC ANTIGENS
#4261Modified cells and methods of therapy
#4262Methods for therapeutic administration of messenger ribonucleic acid drugs
#4263Pharmaceutical composition for preventing or treating cancer comprising KSP inhibitor and mitosis inhibitor
#4264METHODS OF TREATING SCHIZOPHRENIA AND OTHER NEUROPSYCHIATRIC DISORDERS
#4265Compositions and methods for organ specific delivery of nucleic acids
#4266METHODS AND COMPOSITIONS FOR LOCALIZED AGENT DELIVERY
#4267Methods of genetic mediated engineering of RNAi models
#4268ANTI-REFLECTIVE ARTICLES WITH NANOSILICA-BASED COATINGS
#4269Exonic splicing enhancers and exonic splicing silencers
#4270METHOD FOR DETERMINING DECREASE IN FUNCTIONS OF HIPPOCAMPUS BY USING CORRELATION BETWEEN MICRO RNA AND NMDA RECEPTOR, METHOD FOR INHIBITING DECREASE IN FUNCTIONS, AND METHOD FOR SCREENING FOR INHIBITORS OF DECREASE IN FUNCTIONS
#4271METHODS FOR TREATING SPINAL CORD INJURY
#4272DOWN-REGULATING GENE EXPRESSION IN INSECT PLANTS
#4273Composition for editing flavonoid biosynthetic gene by using CRISPR/Cas9 system, and use thereof
#4274TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#4275Oligonucleotide comprising an inosine for treating DMD
#4276SYSTEMS AND METHODS RELATED TO OLIGONUCLEOTIDE BUFFERS
#4277COMBINATION THERAPIES COMPRISING C/EBP ALPHA SARNA
#4278GENOME ENGINEERING PRIMARY MONOCYTES
#4279MICRORNA INHIBITORS FOR USE IN TREATING METABOLIC DISEASES
#4280Nucleic acid molecules and uses thereof
#4281iRNA AGENTS WITH BIOCLEAVABLE TETHERS
#4282Structurally designed shRNAs
#4283SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#4284OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#4285Systems and methods for the treatment of hemoglobinopathies
#4286MIR-3132 UPREGULATION OF THE TRAIL PATHWAY AND APOPTOTIC ACTIVITY IN CANCER CELLS
#4287LINKAGE MODIFIED OLIGOMERIC COMPOUNDS
#4288Short/small hairpin RNA molecules
#4289Compositions and methods for gene editing by targeting transferrin
#4290IDENTIFICATION AND TARGETED MODULATION OF GENE SIGNALING NETWORKS
#4291Single-stranded oligonucleotide
#4292Artificially-manipulated neovascularization regulatory system
#4293EPITOPE OF EPB41L5, AND MONOCLONAL ANTIBODY
#4294Compounds and methods for increasing STMN2 expression
#4295COMBINATION THERAPIES FOR INNER EAR SENSORY HAIR CELL REGENERATION/REPLACEMENT
#4296METHODS OF TREATING DISORDERS
#4297RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#4298Antisense oligonucleotides and their use for treating Pendred syndrome
#4299Composition and methods of RNAi prophylactics and therapeutics for treatment of severe acute respiratory infection caused by 2019 novel coronavirus (2019-nCoV)
#4300Factor XII (Hageman Factor) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), and Kininogen 1 (KNG1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#4301tRNA/pre-miRNA compositions and use in treating cancer
#4302Polynucleotide and method for controlling insect infestation
#4303Polynucleotide and method used for controlling insect invasion
#4304Antisense oligonucleotides to restore dysferlin protein expression in dysferlinopathy patient cells
#4305Electrochemical biosensor
#4306METHOD OF PRODUCING CAR-T CELLS, NUCLEIC ACID-INTRODUCING CARRIER AND KIT
#4307Recombinant polypeptide production method
#4308Methods for expressing proteins in axons
#4309NEUTRAL LIPOSOMES CONTAINING BIOLOGICALLY ACTIVE AGENTS
#4310Systems and methods for determining effects of therapies and genetic variation on polyadenylation site selection
#4311System and Method for the Universal Destruction of Cancer Cells without Toxicity
#4312ENGINEERED CELLS WITH MODIFIED HOST CELL PROTEIN PROFILES
#4313USING MICRORNAS TO CONTROL ACTIVATION STATUS OF HEPATIC STELLATE CELLS AND TO PREVENT FIBROSIS IN PROGRESSIVE LIVER DISEASES
#4314BETA CATENIN NUCLEIC ACID INHIBITOR MOLECULE
#4315RNAi Agents And Compositions for Inhibiting Expression of Angiopoietin-Like 3 (ANGPTL3), And Methods Of Use
#4316Oligonucleotide Conjugates
#4317Bioactive renal cells
#4318Treatment of ophthalmic conditions with son of Sevenless 2 (SOS2) inhibitors
#4319COMPOSITIONS, SYSTEMS, AND METHODS FOR BASE DIVERSIFICATION
#4320Chemically modified single-stranded RNA-editing oligonucleotides
#4321PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING CANCER, CONTAINING CD300C EXPRESSION INHIBITOR OR ACTIVITY INHIBITOR
#4322Modified RNA agents with reduced off-target effect
#4323Compositions and methods for improving strand biased
#4324MicroRNAs as therapeutic targets for ischemic stroke
#4325Chimeric RNA-driven genomic rearrangement in mammalian cells
#4326Selective antisense compounds and uses thereof
#4327Staufen1 regulating agents and associated methods
#4328Suppression of shade avoidance response in plants
#4329Personalized cells, tissues, and organs for transplantation from a humanized, bespoke, designated-pathogen free, (non-human) donor and methods and products relating to same
#4330Synergistic genome-nonintegrating reprogramming by microRNAs and transcription factors
#4331EXTRACELLULAR VESICLES LOADED WITH AN EXOGENOUS MOLECULE
#4332Enhanced placental stem cells and uses thereof
#4333PRODUCING RECOMBINANT PROTEINS WITH REDUCED LEVELS OF HOST CELL PROTEINS
#4334Gene therapy for AADC deficiency
#4335General and direct method for preparing oligonucleotide-functionalized metal-organic framework nanoparticles
#4336Cationic amphiphilic polymers for codelivery of hydrophobic agents and nucleic acids
#4337METHODS OF SUPPORTING WEIGHT MAINTENANCE BY DECREASING THE ACTIVITY OF FAM46A
#4338Compositions and methods for the treatment of expanded repeat-associated disorders
#4339METHODS OF EVALUATING TREATMENT OUTCOME IN HIGH GRADE SEROUS OVARIAN CANCER
#4340Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#4341COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
#4342PLANT REGULATORY ELEMENTS AND USES THEREOF
#4343Plant regulatory elements and uses thereof
#4344RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#4345OLIGONUCLEOTIDES FOR CONTROLLING TAU SPLICING, AND USES THEREOF
#4346Micro-RNAS and compositions comprising same for the treatment and diagnosis of serotonin-, adrenalin-, noradrenalin-, glutamate-, and corticotropin-releasing hormone- associated medical conditions
#4347RIG-I Agonists and Methods of Using Same
#4348BIODEGRADABLE AND CLINICALLY-COMPATIBLE NANOPARTICLES AS DRUG DELIVERY CARRIERS
#4349COMPOSITIONS AND METHODS FOR CONTROLLING LEPTINOTARSA
#4350Programmable conditional SIRNAS and uses thereof
#4351Targeted Self-Assembly of Functionalized Carbon Nanotubes on Tumors
#4352Methods of reducing virus molecule levels
#4353Stereospecific linkages in RNA editing oligonucleotides
#4354Compositions for Modulating C9ORF72 Expression
#4355Methods and systems of molecular recording by CRISPR-Cas system
#4356Method for stabilizing nucleic acid nanostructures
#4357Expanding the chemical substrates for genetic code reprogramming
#4358NOVEL TARGET FOR ANTI-CANCER AND IMMUNE-ENHANCING
#4359METHODS AND COMPOSITIONS TO STIMULATE RETINAL REGENERATION
#4360COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION OF GENE THERAPY VECTORS AND FOR REMOVING OR REDUCING IMMUNOGLOBULINS
#4361Mesenchymal stem cell and use thereof for treatment of muscle injury and muscle-associated diseases
#4362Targeted replacement of endogenous T cell receptors
#4363ANTI-BCMA CAR-T-CELLS FOR PLASMA CELL DEPLETION
#4364Oligonucleotide compositions and methods thereof
#4365LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#4366DRUG-LOADED TISSUE ADHESIVE FILM AND PREPARATION METHOD THEREFOR
#4367Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#4368MODIFIED AAV CONSTRUCTS AND USES THEREOF
#4369POLYNUCLEOTIDE AGENTS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12) AND METHODS OF USE THEREOF
#4370COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANESTHESIA-INDUCED NEUROTOXICITY
#4371Compositions and Methods for Lactate Dehydrogenase (LDHA) Gene Editing
#4372Methods of treating porphyria
#4373CRISPR/CAS9 SYSTEMS, AND METHODS OF USE THEREOF
#4374Von Willebrand Factor (VWF)-targeting agents and methods of using the same
#4375ANTISENSE NUCLEIC ACIDS
#4376METHODS FOR REACTIVATING GENES ON THE INACTIVE X CHROMOSOME
#4377SLC2A1 LNCRNA AS A BIOLOGIC AND RELATED TREATMENTS AND METHODS
#4378LNA BASED NANODEVICE
#4379GENE-DRIVE IN DNA VIRUSES
#4380Incorporation of unnatural nucleotides and methods thereof
#4381PHARMACEUTICAL COMPOSITIONS FOR TREATMENT OF MICRORNA RELATED DISEASES
#4382EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#4383NOVEL LIPID FORMULATIONS FOR NUCLEIC ACID DELIVERY
#4384Polynucleotide and method for controlling insect invasion
#4385COMPOSITIONS FOR DELIVERY OF CARGO TO CELLS
#4386ENHANCED OLIGONUCLEOTIDES FOR INHIBITING SCN9A EXPRESSION
#4387Peptide docking vehicle for targeted nucleic acid delivery
#4388COMPOSITIONS FOR MODULATING EXPRESSION OF C9ORF72 ANTISENSE TRANSCRIPT
#4389Nucleic acid loaded extracellular vesicles
#4390Targeting PAX2 for the treatment of breast cancer
#4391Treatments of non-alcoholic steatohepatitis (NASH)
#4392REPEAT RNA AS BIOMARKERS OF TUMOR IMMUNE RESPONSE
#4393CRISPR DOUBLE NICKASE BASED AMPLIFICATION COMPOSITIONS, SYSTEMS, AND METHODS
#4394VIRAL DELIVERY OF RNA UTILIZING SELF-CLEAVING RIBOZYMES AND CRISPR-BASED APPLICATIONS THEREOF
#4395Methods and compositions for inhibiting detoxification response
#4396Non-liposomal systems for nucleic acid delivery
#4397Programmable and portable CRISPR-Cas transcriptional activation in bacteria
#4398METHOD FOR EFFICIENT EXON (44) SKIPPING IN DUCHENNE MUSCULAR DYSTROPHY AND ASSOCIATED MEANS
#4399RNA-INTERFERENCE-INDUCING NUCLEIC ACID MOLECULE ABLE TO PENETRATE INTO CELLS, AND USE THEREFOR
#4400MYOCARDIAL DYSFUNCTION THERAPEUTIC AGENT
#4401INHIBITION OF FOLLISTATIN
#4402METHODS AND COMPOSITIONS FOR THE MAKING AND USING OF GUIDE NUCLEIC ACIDS
#4403Recruitment of DNA polymerase for templated editing
#4404Genetically-modified cells comprising a modified human T cell receptor alpha constant region gene
#4405Method of reducing expression of DUX4 in a muscle cell by administering an anti-transferrin receptor antibody linked to an oligonucleotide targeting DUX4
#4406RECEPTOR INHIBITION BY PHOSPHATASE RECRUITMENT
#4407Isolation of novel AAV's and uses thereof
#4408Senile dementia treatment formulation and application thereof
#4409ANTIBACTERIAL PHAGE, THERAPEUTIC COMPOSITION, BACTERICIDAL AGENT, FOOD, BACTERIA IDENTIFICATION KIT, THERAPEUTIC COMPOSITION MANUFACTURING METHOD, BACTERIA ELIMINATION METHOD, BACTERIA IDENTIFICATION METHOD, AND ANIMAL THERAPEUTIC METHOD
#4410MICROENCAPSULATED MODIFIED POLYNUCLEOTIDE COMPOSITIONS AND METHODS
#4411METHODS FOR DETERMINING THE PRESENCE OR RISK OF DEVELOPING FACIOSCAPULOHUMERAL DYSTROPHY (FSHD)
#4412KIT FOR REPARING FBN1T7498C MUTATION, COMBINATION FOR MAKING AND REPAIRING MUTATION, AND METHOD OF REPAIRING THEREOF
#4413Gene editing method using virus
#4414METHOD FOR INCREASING THE YIELD OF MICROALGAE AND PRODUCTS PRODUCED THEREBY, AN ALTERED CAM1 GENE AND POLYPEPTIDE, AND A NOVEL CHLAMYDOMONAS SP.
#4415RNA targeting of mutations via suppressor tRNAs and deaminases
#4416Method for knocking out N-myristoyltransferase (NMT) gene from
#4417Compositions and methods for treating and preventing muscular disorders and dystrophies, steroid side effects, and inflammation
#4418Methods and formulations for the treatment of obesity and obesity-related metabolic diseases
#4419ANTIFIBROTIC AGENT AND BIOMARKER FOR FIBROSIS
#4420ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF
#4421NOVEL CRISPR-ASSOCIATED SYSTEMS AND COMPONENTS
#4422MAD nucleases
#4423Use of Syncytin for Targeting Drug and Gene Delivery to Lung Tissue
#4424ANTI-IL-23 ANTIBODIES
#4425MODULATED CAS-INHIBITORS
#4426RECOMBINANT NEWCASTLE DISEASE VIRUSES AND USES THEREOF FOR THE PREVENTION OF RSV DISEASE OR HUMAN METAPNEUMOVIRUS DISEASE
#4427Antisense nucleic acids
#4428OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#4429BACTERIAL DELIVERY VEHICLES FOR IN VIVO DELIVERY OF A DNA PAYLOAD
#4430FUNCTIONAL NUCLEIC ACID HAVING NUCLEOSIDE ANALOG DRUG INTEGRATED INTO SKELETON, DERIVATIVE AND USE THEREOF
#4431Liposomal-gold nanoparticles for drug delivery into the brain
#4432SEQUENTIAL PAIRED-END SEQUENCING
#4433System for DNA editing and uses thereof
#4434COMPOSITIONS AND METHODS OF USE OF ARC CAPSIDS
#4435AAV vectors for retinal and CNS gene therapy
#4436CRISPR INTERFERENCE BASED HTT ALLELIC SUPPRESSION AND TREATMENT OF HUNTINGTON DISEASE
#4437Creation of herbicide resistant gene and use thereof
#4438Expression from transposon-based vectors and uses
#4439Composition for preventing or treating neurodegenerative disease
#4440Targeting ligands for therapeutic compounds
#4441COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF FACTOR V
#4442S-ANTIGEN TRANSPORT INHIBITING OLIGONUCLEOTIDE POLYMERS AND METHODS
#4443Programmed cell death 1 ligand 1 (PD-L1) iRNA compositions and methods of use thereof
#4444Combination treatment for cystic fibrosis
#4445METHODS OF MODULATING ANK1
#4446DNA-guided gene editing and regulation
#4447Method for regulating gene expression
#4448ENHANCED REPROGRAMMING OF SOMATIC CELLS
#4449COMPOSITIONS AND METHODS FOR MODULATING MONOCYTE AND MACROPHAGE INFLAMMATORY PHENOTYPES AND IMMUNOTHERAPY USES THEREOF
#4450SINGLE-STRANDED NUCLEIC ACID MOLECULE, AND PRODUCTION METHOD THEREFOR
#4451COMPOSITIONS AND METHODS FOR GENE EDITING FOR HEMOPHILIA A
#4452Compositions and methods of treating muscle atrophy and myotonic dystrophy
#4453Modified factor VII polypeptides for subcutaneous administration and on-demand treatment
#4454IPSC-DERIVED SECRETOME COMPOSITIONS, AND RELATED SYSTEMS AND METHODS
#4455CYTOBIOLOGICS AND THERAPEUTIC USES THEREOF
#4456C/EBP ALPHA SARNA COMPOSITIONS AND METHODS OF USE
#4457EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
#4458COMPOSITIONS AND USES THEREOF
#4459Control of plant pests using RNA molecules
#4460Transgene cassettes designed to express a human MECP2 gene
#4461Compositions and methods for inhibiting gene expression of Hif2alpha
#4462Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#4463Exon skipping compositions for treating muscular dystrophy
#4464ANTI-ARID3A TREATMENTS FOR INFLAMMATORY DISORDERS
#4465Modulating SYNGAP
#4466Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA
#4467MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
#4468COMPOSITIONS AND METHODS FOR IMPROVING THE EFFICACY OF CAS9-BASED KNOCK-IN STRATEGIES
#4469Methods and compositions for studying cell evolution
#4470MODULATORS OF ENaC EXPRESSION
#4471Method for treating cancer by disabling-BRCA1/FANCM interaction
#4472Systems and methods for gene modification
#4473RECOMBINANT AAVS HAVING USEFUL TRANSCYTOSIS PROPERTIES
#4474Enhanced immune effector cells and use thereof
#4475PLATELETS LOADED WITH mRNA
#4476Method of assessing activity of recombinant antigen receptors
#4477Nucleic acid-polypeptide compositions and uses thereof
#4478ANTISENSE NUCLEIC ACIDS
#4479Skin-permeating carrier containing nucleic acid complex and use thereof
#4480COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#4481POROUS SILICON MATERIALS COMPRISING A METAL SILICATE FOR DELIVERY OF THERAPEUTIC AGENTS
#4482METHODS AND COMPOSITIONS TO IDENTIFY NOVEL CRISPR SYSTEMS
#4483Genomic safe harbors for genetic therapies in human stem cells and engineered nanoparticles to provide targeted genetic therapies
#4484Increasing plant oil content by altering a negative regulator of acetyl-CoA carboxylase
#4485bZIP transcription factors regulate conversion of nicotine to nornicotine
#4486Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#4487Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#4488Targeting Mirnas for Exosomal Delivery or Cellular Retention
#4489COMPOSITIONS AND METHODS FOR TARGETING GLYPICAN-2 IN THE TREATMENT OF CANCER
#4490Recruitment methods and compounds, compositions and systems for recruitment
#4491COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)
#4492METHODS OF MODULATING ANTISENSE ACTIVITY
#4493Compositions and methods for modulating gene expression
#4494Polyanionic acids to improve recovery and minimize system loss
#4495MAD nucleases
#4496Use of SRSF3 agents for the treatment and/or prevention of neurological conditions, cancer, bacterial infections or viral infections
#4497Compounds for use in the treatment of telomere related diseases and/or telomere related medical conditions
#4498EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#4499Conjugated Antisense Compounds for Use in Therapy
#4500METHODS FOR REDUCING C9ORF72 EXPRESSION