109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
MODULATING TRANSCRIPTIONAL CONDENSATES
#1502METHODS FOR ENHANCING UTROPHIN PRODUCTION VIA INHIBITION OF MICRORNA
#1503MODIFIED DOUBLE-STRANDED DONOR TEMPLATES
#1504Fusion Proteins for CRISPR-based Transcriptional Repression
#1505COMPOSITIONS AND METHODS FOR THE GENERATION OF NEURONS AND USES THEREOF
#1506Complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide
#1507LIPIDS FOR USE IN LIPID NANOPARTICLE FORMULATIONS
#1508METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY TARGETING AXL SIGNALING
#1509ASSESSING RISK FOR COLORECTAL ADENOMA RECURRENCE BY NONINVASIVE MEANS
#1510COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING
#1511KLF11 siRNA For Treatment Of Diabetes And Obesity
#1512COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION
#1513SMALL INTERFERING RNA TARGETING C3 AND USES THEREOF
#1514METHOD FOR MODULATING UNPRODUCTIVE ALTERNATIVE SPLICING
#1515UNA AMIDITES AND USES THEREOF
#1516iRNA Compositions and Methods for Silencing Filamin A (FLNA)
#1517METHODS AND COMPOSITIONS FOR TREATING CHRONIC LIVER DISEASE AND HEPATOCELLULAR CARCINOMA
#1518Combination of Antisense Oligomers
#1519COMPOUNDS FOR MODULATING UNC13A EXPRESSION
#1520MICRORNA-134 INHIBITORS
#1521COMPOSITIONS AND METHODS USEFUL FOR THE TREATMENT OF BONE MARROW FAILURE DISEASES ASSOCIATED WITH RIBOSOMOPATHIES
#1522COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION
#1523COMPOUNDS AND METHODS FOR REDUCING APP EXPRESSION
#1524OLIGONUCLEOTIDES FOR HTT-1A MODULATION
#1525Chemically Modified Small Activating RNA
#1526MICRORNA 195 COMPOSITIONS AND METHODS FOR TREATING COGNITIVE IMPAIRMENT
#1527COMPOSITION COMPRISING MIR 145 INHIBITOR AS ACTIVE INGREDIENT FOR TREATMENT OF MYOCARDIAL INFARCTION
#1528COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)
#1529METHODS FOR CONTROLLING MERISTEM SIZE FOR CROP IMPROVEMENT
#1530MICROPEPTIDES AND USE OF SAME FOR MODULATING GENE EXPRESSION
#1531INHIBITORS OF DNA-DEPENDENT PROTEIN KINASE AND COMPOSITIONS AND USES THEREOF
#1532NON-CODING RNA PROTECTING AGAINST HEART FAILURE
#1533CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE
#1534AGENT FOR USE IN THE TREATMENT OF GLIOMA
#1535COMPOSITION FOR ALLEVIATING HAIR GRAYING, PROMOTING HAIR GROWTH AND/OR PREVENTING OR ALLEVIATING HAIR LOSS, COMPRISING DOUBLE-STRANDED MIRNA AS ACTIVE INGREDIENT
#1536NOVEL REDOX-BASED THERAPEUTIC APPROACH FOR TREATMENT OF CANCER
#1537LIPID NANOPARTICLES AND METHOD FOR PREPARING SAME
#1538METHODS OF PLACING LOCKED NUCLEIC ACIDS IN SMALL INTERFERING RNA STRANDS
#1539CELL-BASED ASSAY FOR QUANTIFYING THE POTENCY AND EFFICACY OF CANNABINOIDS AND/OR TERPENOIDS, AND METHODS OF USE THEREOF
#1540RNA-guided nucleases and active fragments and variants thereof and methods of use
#1541RAPAMYCIN RESISTANT CELLS
#1542METHOD FOR IMPROVING GENETIC ENGINEERING OF ADOPTIVE CELL THERAPIES
#1543Means and Methods for Improved Regeneration
#1544Organelle genome modification using polynucleotide guided endonuclease
#1545Selective Antisense Compounds and Uses Thereof
#1546SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#1547Oligonucleotides for Modulating Apolipoprotein E4 Expression
#1548COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B VIRUS INFECTION
#1549Methods and Compositions for Treatment of Polycystic Kidney Disease
#1550COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1551INSULIN-LIKE GROWTH FACTOR BINDING PROTEIN, ACID LABILE SUBUNIT (IGFALS) AND INSULIN-LIKE GROWTH FACTOR 1 (IGF-1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1552NOVEL THERAPEUTIC AGENT FOR SEPTICEMIA, AND A METHOD FOR SCREENING FOR SAME
#1553AGENTS, COMPOSITIONS, AND METHODS FOR THE TREATMENT OF HYPOXIA AND ISCHEMIA-RELATED DISORDERS
#1554USE OF MIRNA-485 INHIBITORS FOR TREATING DISEASES OR DISORDERS ASSOCIATED WITH ABNORMAL NLRP3 EXPRESSION
#1555SELECTIVE DELIVERY OF OLIGONUCLEOTIDES TO GLIAL CELLS
#1556ATXN2 IRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING ATXN2-ASSOCIATED NEURODEGENERATIVE DISEASES
#1557ANTISENSE OLIGONUCLEOTIDES FOR INCREASING SHANK3 EXPRESSION
#1558RNA-ONLY DERIVED ORTHOMYXOVIRUSES AND ASSOCIATED VECTORS AND USES THEREOF
#1559Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of use thereof to target dystrophin and to treat Duchenne muscular dystrophy
#1560GLP-1 RECEPTOR LIGAND MOIETY CONJUGATED OLIGONUCLEOTIDES AND USES THEREOF
#1561CARBOHYDRATE CONJUGATES FOR THE DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#1562BRANCHED OLIGONUCLEOTIDES
#1563COMPOSITIONS AND METHODS FOR INCREASING THE SERUM HALF-LIFE OF A THERAPEUTIC AGENT TARGETING COMPLEMENT C5
#1564METHODS FOR DIAGNOSIS AND TREATMENT OF TYPE 1 DIABETES
#1565CONTROL OF PLANT PESTS USING RNA MOLECULES
#1566METHOD FOR MODIFYING TARGET SITE IN GENOME OF EUKARYOTIC CELL, AND METHOD FOR DETECTING PRESENCE OR ABSENCE OF NUCLEIC ACID SEQUENCE TO BE DETECTED AT TARGET SITE
#1567NOVEL PROCESSES FOR THE PRODUCTION OF OLIGONUCLEOTIDES
#1568COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM
#1569COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#1570Allele-specific silencing therapy for DFNA21 using antisense oligonucleotides
#1571METHOD FOR SYNTHESIS OF LINKAGE MODIFIED OLIGOMERIC COMPOUNDS
#1572TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS
#1573TREATMENT OF MTRES1 RELATED DISEASES AND DISORDERS
#1574TREATMENT OF PLIN1 RELATED DISEASES AND DISORDERS
#1575COMPOSITIONS AND METHODS OF USE FOR MUTATED HOTAIR IN THE TREATMENT OF CANCERS
#1576RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#1577OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION
#1578Compounds and Methods for Modulating Splicing of Pre-MRNA
#1579LIPID CONJUGATION FOR TARGETING NEURONS OF THE CENTRAL NERVOUS SYSTEM
#1580Antisense Oligomer
#1581OLIGONUCLEOTIDES
#1582NANO COMPLEX FOR TARGETED REPAIRING OF NEUROVASCULAR LESION, AND PREPARATION AND USE THEREOF
#1583COMPOSITIONS AND METHODS FOR MULTIPLEXED QUANTITATIVE ANALYSIS OF CELL LINEAGES
#1584PSEUDOTYPED VIRAL PARTICLES, COMPOSITIONS COMPRISING THE SAME, AND USES THEREOF
#1585ENGRAFTABLE CELL-BASED IMMUNOTHERAPY FOR LONG-TERM DELIVERY OF THERAPEUTIC PROTEINS
#1586Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide
#1587COMPOSITIONS AND METHODS FOR CELL TYPE-SPECIFIC GENE EXPRESSION IN THE INNER EAR
#1588TREATMENT OF PRIMARY CILIARY DYSKINESIA WITH SYNTHETIC MESSENGER RNA
#1589COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#1590COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#1591PRECIPITATION SUPPRESSING AGENT
#1592GENETICALLY MODIFIED NK CELLS AND USES THEREOF
#1593Compounds and Methods for Modulating GFAP
#1594FORMULATIONS FOR ORAL DELIVERY OF NUCLEIC ACIDS
#1595NEPHROTOXICITY REDUCING AGENT
#1596Use of micro-ribonucleic acid (miRNA) to diagnose transplant rejection and tolerance of immunosuppression therapy
#1597METHODS FOR PRODUCTION AND QUANTIFICATION OF UNIQUE MOLECULAR IDENTIFIER-LABELED BEADS
#1598PEPTIDE NUCLEIC ACIDS FOR SPATIOTEMPORAL CONTROL OF CRISPR-CAS BINDING
#1599VECTOR-FREE DELIVERY OF GENE EDITING PROTEINS AND COMPOSITIONS TO CELLS AND TISSUES
#1600Conjugated antisense compounds and their use
#1601HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#1602Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors
#1603RECRUITMENT METHODS AND COMPOUNDS, COMPOSITIONS AND SYSTEMS FOR RECRUITMENT
#1604DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#1605COMPOSITIONS AND METHODS FOR THE PREVENTION AND TREATMENT OF HEMOGLOBINOPATHIES
#1606Engineered Guide RNAs and Polynucleotides
#1607LIGAND-BINDING NUCLEIC ACID COMPLEX
#1608COMPOUNDS FOR REDUCING PTBP1 EXPRESSION
#1609FOLLICULIN iRNA COMPOSITIONS AND METHODS THEREOF
#1610RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#1611METHODS FOR CONTROLLING MERISTEM SIZE FOR CROP IMPROVEMENT
#1612CRISPR/CAS9-BASED REPRESSORS FOR SILENCING GENE TARGETS IN VIVO AND METHODS OF USE
#1613METHOD FOR IMMORTALISING VESICLE-SECRETING CELLS
#1614CD71 BINDING FIBRONECTIN TYPE III DOMAINS
#1615siRNA DELIVERY VECTOR
#1616PLANT REGULATORY ELEMENTS AND USES THEREOF
#1617LPA INHIBITOR AND USE THEREOF
#1618Engineered Guide RNAs and Polynucleotides
#1619METHODS AND COMPOSITIONS FOR MODULATING STING SIGNALING AND INNATE IMMUNE RESPONSES
#1620Asymmetric Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#1621COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1622COMPOSITION COMPRISING AN RNA THERAPEUTIC TARGETING FAT10 AND USES OF SAME FOR TREATING DISORDERS CHARACTERIZED BY ABNORMAL LIPID ACCUMULATION
#1623OLIGONUCLEOTIDES AND COMPOSITIONS THEREOF FOR NEUROMUSCULAR DISORDERS
#1624KRAB-Containing Zinc Finger Protein And Cancer
#1625MIRNA INHIBITORS FOR PREVENTING AND TREATING ANEURYSMS, HYPERTENSION, ARDS AND OTHER DISEASES ASSOCIATED WITH ENDOTHELIAL DYSFUNCTION
#1626Chemically modified single-stranded rna-editing oligonucleotides
#1627LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF INFLAMMATORY DISEASES
#1628ENGINEERED PROTEINS AND METHODS OF USE THEREOF
#1629METHODS AND COMPOSITIONS FOR CELL REPROGRAMMING
#1630METHODS AND COMPOSITIONS FOR TREATING OCULAR DISEASES AND DISORDERS
#1631EXTRACELLULAR VESICLE-ENRICHED SECRETOME COMPOSITION DERIVED FROM INDUCED PLURIPOTENT STEM CELL DERIVED-MICROGLIA AND METHODS OF USE THEREOF
#1632METHODS AND COMPOSITIONS FOR TAU REDUCTION GENE THERAPY
#1633Use Of Citicoline In Regulating Respiratory Chain Function Related Protein Level And Preparing Drug For Preventing And Treating Respiratory Chain Dysfunction
#1634COLORECTAL CANCER DETECTION KIT OR DEVICE, AND DETECTION METHOD
#1635TREATMENT OF SCHIZOPHRENIA AND BIPOLAR DISORDER
#1636COMPOSITIONS AND METHODS FOR PRODUCING CIRCULAR POLYRIBONUCLEOTIDES
#1637ANIMAL PREPARATION METHOD
#1638METHODS OF ALTERING GENE EXPRESSION BY PERTURBING TRANSCRIPTION FACTOR MULTIMERS THAT STRUCTURE REGULATORY LOOPS
#1639METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#1640Use Of LncRNA DCRT As Drug And Its Drug For Treating Cardiovascular Diseases, Screening Method, And Preparation Method Thereof
#1641Methods and Compositions for Adar-Mediated Editing
#1642NUCLEIC ACID MOLECULE TARGETING MUTATION SITE OF CYP4V2 GENE AND USE THEREOF
#1643COMPOSITION FOR TREATING METASTATIC SOLID CANCER, COMPRISING TSG6 INHIBITOR
#1644EXPRESSION-INDUCING AGENT FOR CLASS I GLUCOSE TRANSPORTER (GLUT), AND MEDICINAL COMPOSITION AND FOOD COMPOSITION USING SAME
#1645USE OF A FUSION PROTEIN FOR INDUCING GENETIC MODIFICATIONS BY TARGETED MEIOTIC RECOMBINATION
#1646TIM-3 MODULATES ANTI-TUMOR IMMUNITY BY REGULATING INFLAMMASOME ACTIVATION
#1647MODULAR LIPID COMPOUNDS AND TWO- TO THREE-COMPONENT LIPID NANOPARTICLE COMPOSITIONS
#1648SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
#1649SYSTEMS AND METHODS FOR REGULATING TARGET GENES
#1650Methods and Compositions for Determining pH
#1651PRODUCTS AND METHODS FOR TREATMENT OF DYSTROPHIN-BASED MYOPATHIES USING CRISPR-CAS9 TO CORRECT DMD EXON DUPLICATIONS
#1652BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1653Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#1654COMPOSITIONS AND METHODS OF TARGETING THE PAX6 SIGNALING PATHWAY TO REDUCE FORMATION OF AMYLOID BETA PLAQUES AND NEUROFIBRILLARY TANGLES
#1655ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES
#1656MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1657COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#1658SIRNAS TARGETING SLC10A1 TRANSCRIPTS, COMPOSITIONS AND USES THEREOF
#1659SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION FACTOR 6 (STAT6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1660COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF FRATAXIN (FXN)
#1661METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#1662EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
#1663MODIFIED NUCLEIC ACID INHIBITING MICRO RNA, AND USE THEREOF
#1664COMPOSITIONS AND METHODS FOR MODULATING SECRETED FRIZZLED RECEPTOR PROTEIN 1 (SFRP1) GENE EXPRESSION
#1665SINGLE-COMPONENT NEAR-INFRARED OPTOGENETIC SYSTEMS FOR GENE TRANSCRIPTION REGULATION
#1666Targeting Nuclear Speckles and DNA Speckle Association
#1667RABIES VIRAL GLYCOPROTEIN COMPOSITIONS AND METHODS OF USE
#1668GENE THERAPY FOR WET AGE-RELATED MACULAR DEGENERATION USING IPSC-DERIVED CELLS AS VECTORS
#1669CARBOHYDRATE CONJUGATED RNA AGENTS AND PROCESS FOR THEIR PREPARATION
#1670Compositions and methods for organ-protective expression and modulation of coding ribonucleic acids
#1671Nanomaterials comprising triols
#1672FATTY ACID CONJUGATES OF NUCLEIC ACIDS
#1673RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#1674CONSTRUCTS AND METHODS FOR PREPARING CIRCULAR RNA
#1675NOVEL lncRNA CONTROLLING CARDIAC FIBROSIS
#1676METHOD FOR DESIGNING OLIGONUCLEOTIDE HAVING REDUCED CENTRAL TOXICITY
#1677CRISPR/CAS SYSTEM AND METHOD FOR GENOME EDITING AND MODULATING TRANSCRIPTION
#1678miRNA Switches for RNA-Triggered Control of RNA Interference
#1679CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#1680COMPOSITIONS AND METHODS FOR MODULATING GENE EXPRESSION
#1681OLIGONUCLEOTIDE AND TARGET RNA SITE-SPECIFIC EDITING METHOD
#1682POLYNUCLEOTIDE CONSTRUCTS
#1683CATIONIC LIPIDS FOR NUCLEIC ACID DELIVERY AND PREPARATION THEREOF
#1684TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#1685IONIZABLE LIPID COMPOUNDS
#1686COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#1687COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#1688MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#1689Heteronucleic acid containing scpBNA or AmNA
#1690HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1691NEUROPROTECTIVE MOLECULES AND METHODS OF TREATING NEUROLOGICAL DISORDERS AND INDUCING STRESS GRANULES
#1692RAAV-BASED COMPOSITIONS AND METHODS
#1693THERAPY FOR TREATMENT OF PRADER-WILLI SYNDROME
#1694SIRNA CONSTRUCTS FOR INHIBITING GENE EXPRESSION IN TARGETED CANCER CELLS
#1695MULTITARGETING RNA COMPOSITIONS
#1696PREVENTION OR TREATMENT OF MYOPATHY USING MIR-33B INHIBITOR
#1697POLYANIONIC ACIDS TO IMPROVE RECOVERY AND MINIMIZE SYSTEM LOSS
#1698Muscle targeting complexes and uses thereof for treating myotonic dystrophy
#1699COMPOSITIONS AND METHODS FOR MODULATION OF SMN2 SPLICING IN A SUBJECT
#1700MODIFIED OLIGOMERIC COMPOUNDS COMPRISING TRICYCLO-DNA NUCLEOSIDES AND USES THEREOF
#1701PHARMACEUTICAL COMPOSITION FOR TREATMENT OF PANCREATIC CANCER AND BILE DUCT CANCER
#1702IN-SITU CRYO-IMMUNE ENGINEERING FOR CANCER IMMUNOTHERAPY
#1703METHODS OF TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS
#1704METHODS FOR ANALYZING NUCLEIC ACID SEQUENCES
#1705COMPOSITIONS AND METHODS FOR RECOMBINANT PARVOVIRUS PRODUCTION
#1706Compositions for Inhibiting Growth of Targeted Cells
#1707Multitargeting RNA Immunotherapy Compositions
#1708MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF NERVOUS SYSTEM DYSFUNCTION
#1709NUCLEIC ACID MOLECULES FOR PSEUDOURIDYLATION
#1710COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#1711SPLICE-SWITCHING OLIGONUCLEOTIDES AND METHODS OF USE
#1712NUCLEIC ACID DELIVERY SYSTEM AND APPLICATION THEREOF
#1713CHIRAL CONTROL
#1714siRNA AND USE THEREOF
#1715tRNA, AMINOACYL tRNA, REAGENT FOR POLYPEPTIDE SYNTHESIS, INTRODUCTION METHOD OF UNNATURAL AMINO ACID, PRODUCTION METHOD OF POLYPEPTIDE, PRODUCTION METHOD OF NUCLEIC ACID DISPLAY LIBRARY, NUCLEIC ACID-POLYPEPTIDE CONJUGATE, AND SCREENING METHOD
#1716MODIFIED NUCLEIC ACIDS, HYBRID GUIDE RNAS, AND USES THEREOF
#1717TUNING CRISPR/CAS9 ACTIVITY WITH CHEMICALLY MODIFIED NUCLEOTIDE SUBSTITUTIONS
#1718Compositions and methods for improved malonyl-CoA biosynthesis using 2-stage dynamic metabolic control
#1719VON WILLEBRAND FACTOR (VWF) INHIBITORS
#1720METHODS AND PRODUCTS FOR GENETIC ENGINEERING
#1721Materials and Methods for Treatment of Hemoglobinopathies
#1722NOVEL LIPID COMPOUND AND LIPID NANOPARTICLE COMPOSITION COMPRISING THE SAME
#1723COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#1724MIR200C-EPCAM AXIS REPROGRAMED IMMUNE CELLS FOR ENHANCED ANTI-TUMOR FUNCTION
#1725USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#1726COMPOSITION FOR TREATING OSTEOARTHRITIS
#1727CHLORELLA-BASED PRODUCTION OF EXTRACELLULAR VESICLE-EMBEDDED SMALL RNAs FOR PROPHYLACTIC OR THERAPEUTIC APPLICATIONS
#1728COAGULATION FACTOR V (F5) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1729FORMULATION OF AN ANTISENSE OLIGOMER CONJUGATE
#1730Signal boost cascade assay
#1731OPTIMIZED 2'- MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE
#1732REPROGRAMMING OF NON-NEURONAL CELLS INTO NEURONS AND METHODS AND COMPOSITIONS TO TREAT NEURODEGENERATIVE DISEASES AND DISORDERS
#1733MODULATING APOLIPOPROTEIN (A) EXPRESSION
#1734SMALL ACTIVATING RNA INCREASING SHANK EXPRESSION AND METHOD OF TREATING INTELLECTUAL DISABILITIES AND ASSOCIATED COMORBIDITIES ASSOCIATED WITH SHANK HAPLOINSUFFICIENCY
#1735METHOD OF TREATING BREAST CANCER IN A SUBJECT BY INHIBITING NIP7 AND A PHARMACEUTICAL COMPOSITION COMPRISING A NIP7 INHIBITOR
#1736CHITOSAN-CONTAINING NANOPARTICLES FOR DELIVERY OF POLYNUCLEOTIDES
#1737EXTRACELLULAR VESICLES WITH TARGETING MOIETY
#1738MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA
#1739COMPOSITIONS AND METHODS FOR TARGETED DELIVERY TO CELLS
#1740INHIBITOR OF SUV39H1 HISTONE METHYLTRANSFERASE FOR USE IN CANCER COMBINATION THERAPY
#1741COMPOSITIONS AND METHODS FOR ENHANCING GENE EXPRESSION
#1742Complement component C3 iRNA compositions and methods of use thereof
#1743EXTRACELLULAR VESICLE COMPOSITIONS
#1744INHIBITORY NUCLEIC ACIDS FOR FACTOR H FAMILY PROTEINS
#1745HIGH EFFICIENCY TRANS-SPLICING FOR REPLACEMENT OF TARGETED RNA SEQUENCES IN HUMAN CELLS
#1746METHOD FOR IMPROVING DIABETIC WOUND HEALING USING MIR-200B
#1747COMPOUNDS AND METHODS FOR MODULATING PLP1
#1748OLIGONUCLEOTIDES FOR TREATING EXPANDED REPEAT DISEASES
#1749Linear DNA with Enhanced Resistance Against Exonucleases
#1750TREATING CANCER
#1751PRODUCTS AND METHODS FOR INDUCING EXON 2 SKIPPING OF THE DMD GENE IN TREATING MUSCULAR DYSTROPHY
#1752METHODS, SYSTEMS, AND APPARATUS FOR IDENTIFYING TARGET SEQUENCES FOR CAS ENZYMES OR CRISPR-CAS SYSTEMS FOR TARGET SEQUENCES AND CONVEYING RESULTS THEREOF
#1753COAGULATION FACTOR V (F5) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1754DNA CONSTRUCTS COMPRISING ALTERNATIVE PROMOTERS
#1755REDIRECTING RISC FOR RNA EDITING
#1756PROGRAMMABLE CAS9-RECOMBINASE FUSION PROTEINS AND USES THEREOF
#1757UMBILICAL CORD MESENCHYMAL CELL EXTRACELLULAR VESICLES FOR THE TREATMENT OF OSTEOARTICULAR AND AUTOIMMUNE DISEASES
#1758MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#1759COMPOSITIONS AND METHODS FOR DELIVERY AND EXPRESSION OF SMALL INHIBITORY PEPTIDES AND USE THEREOF
#1760HIGH STEROL-CONTAINING LIPID NANOPARTICLES
#1761ORAL DELIVERY OF OLIGONUCLEOTIDES
#1762COMPOSITION FOR DIAGNOSIS OR TREATMENT OF ANTICANCER DRUG RESISTANCE
#1763FUSION PROTEINS COMPRISING AN INTEIN POLYPEPTIDE AND METHODS OF USE THEREOF
#1764NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE
#1765METHOD AND COMPOSITIONS FOR PREVENTING TUMOR DEVELOPMENT AND METASTASIS
#1766FUNCTIONAL NUCLEIC ACID MOLECULES DIRECTED TO TARGETS FOR NERVOUS SYSTEM DISORDERS
#1767Allogeneic Cartilage Regeneration
#1768NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF A TARGET GENE COMPRISING PHOSPHORODITHIOATE LINKAGES
#1769EXPANDING THE CHEMICAL SUBSTRATES FOR GENETIC CODE REPROGRAMMING
#1770Synthetic Near-Threshold Translational Repressors
#1771RNAi-NANOPARTICLE CONJUGATE, COMPOSITION, AND METHOD OF SYNTHESIS THEREOF
#1772Compositions for Modulating C9ORF72 Expression
#1773PRODUCTS AND METHODS FOR TREATING MUSCULAR DYSTROPHY
#1774COMPOSITIONS AND METHODS USEFUL FOR THE TREATMENT OF H-ABC LEUKODYSTROPHY
#1775GENE THERAPY FOR INFLAMMATORY CONDITIONS
#1776MICROGLIAL GENE SILENCING USING DOUBLE-STRANDED SIRNA
#1777METHODS OF TREATING DUCHENNE MUSCULAR DYSTROPHY USING PEPTIDE-OLIGONUCLEOTIDE CONJUGATES
#1778TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#1779NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#1780SMALL PEPTIDE COMPOSITIONS AND USES THEREOF
#1781ORAL DELIVERY OF NANOPARTICLES FOR KIDNEY DISEASE
#1782SYSTEMS AND METHODS FOR EXOSOME DELIVERY OF MICRORNAS FOR CELLULAR REPROGRAMMING
#1783TISSUE-SPECIFIC NUCLEIC ACID DELIVERY BY MIXED CATIONIC LIPID PARTICLES
#1784TRANSGENE CASSETTES DESIGNED TO EXPRESS A HUMAN MECP2 GENE
#1785DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES
#1786REGULATION OF GENE EXPRESSION THROUGH APTAMER-MODULATED POLYADENYLATION
#1787TREATMENT OF TUMORS WITH MIRNA TARGETING CDK4/CDK6
#1788Tuning cascade assay kinetics via molecular design
#1789COMPOUNDS AND METHODS FOR REDUCING NLRP3 EXPRESSION
#1790COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION
#1791SPINAL MUSCULAR ATROPHY (SMA) TREATMENT VIA TARGETING OF SMN2 SPLICE SITE INHIBITORY SEQUENCES
#1792CONJUGATES OF SIRNA AND ANTISENSE OLIGONUCLEOTIDES (SIRNASO) AND METHODS OF USE IN GENE SILENCING
#1793RNA SILENCING AGENTS AND METHODS OF USE
#1794ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF NEUROLOGICAL DISORDERS
#1795SMAD2 INHIBITION IN BETA CELLS FOR TYPE 2 DIABETES THERAPY
#1796TYPE VI CRISPR ORTHOLOGS AND SYSTEMS
#1797METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES
#1798COMPOSITIONS AND METHODS FOR TREATING SPINAL MUSCULAR ATROPHY
#1799USE OF MICRORNA-146A AND NANOCERIA CONJUGATE TO IMPROVE WOUND HEALING AND PROMOTE TISSUE REGENERATION
#1800MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes