109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
Polymer nanoparticle and DNA nanostructure compositions and methods for non-viral delivery
#1802CATIONIC LIPIDS AND USES THEREOF
#1803NOVEL CRISPR ENZYMES AND SYSTEMS
#1804GENOMIC INSULATOR ELEMENTS AND USES THEREOF
#1805CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#1806SHORT MULTI-REPEAT RNA TARGETING GENE SILENCING
#1807ENHANCED OLIGONUCLEOTIDES FOR INHIBITING RTELl EXPRESSION
#1808OLIGONUCLEOTIDE THERAPEUTICS AND APPLICATION THEREOF
#1809VARIANT RNAi
#1810Non-liposomal systems for nucleic acid delivery
#1811COMPOSITIONS AND METHODS FOR MODULATING SOS GENE EXPRESSIONS
#1812INHIBITION OF FGR REDUCES FIBROSIS
#1813DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS
#1814Methods of Rescuing Stop Codons via Genetic Reassignment with ACE-tRNA
#1815REPROGRAMMING OF CELLS AND USES THEREOF
#1816CALCIUM VOLTAGE-GATED CHANNEL AUXILIARY SUBUNIT GAMMA 1 (CACNG1) BINDING PROTEINS AND CACNG1-MEDIATED DELIVERY TO SKELETAL MUSCLE
#1817ENGINEERED CHIMERIC FUSION PROTEIN COMPOSITIONS AND METHODS OF USE THEREOF
#1818VIRAL EXPRESSION CONSTRUCT COMPRISING A FIBROBLAST GROWTH FACTOR 21 (FGF21) CODING SEQUENCE
#1819STAUFEN1 AGENTS AND ASSOCIATED METHODS
#1820EXTRACELLULAR VESICLES LOADED WITH AT LEAST TWO DIFFERENT NUCLEIC ACIDS
#1821THIN-SHELL POLYMERIC NANOPARTICLES AND USES THEREOF
#1822OPTICAL TRANSMISSION SAMPLE HOLDER AND ANALYSIS, PARTICULARLY FOR HEMOGLOBIN
#1823RNA-Guided Transcriptional Regulation
#1824VECTORS
#1825ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1826DOSING OF siRNA COMPOUNDS TO THE CISTERNA MAGNA
#1827ANTI-C5 ANTIBODY/C5 IRNA CO-FORMULATIONS AND COMBINATION THERAPIES
#1828SMALL INTERFERING RNA TARGETING C3 AND USES THEREOF
#1829ANTISENSE OLIGONUCLEOTIDES THAT BIND TO EXON 51 OF HUMAN DYSTROPHIN PRE-MRNA
#1830DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES
#1831GalNAc compositions for improving siRNA bioavailability
#1832RUNX1 Inhibition for Treatment of Proliferative Vitreoretinopathy and Conditions Associated with Epithelial to Mesenchymal Transition
#1833METHODS FOR MODULATING FMR1 EXPRESSION
#1834COMPOSITIONS OF MODIFIED TREMS AND USES THEREOF
#1835Skeletal Muscle Delivery Platforms and Methods of Use
#1836OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1837COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1838OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1839METHOD FOR SITE-SPECIFIC CONJUGATION OF NUCLEIC ACID TO CRISPR FAMILY PROTEIN, AND CONJUGATE THEREOF AND USE THEREOF
#1840SYSTEM AND METHOD FOR GENOME EDITING BASED ON C2C1 NUCLEASES
#1841Cationic sulfonamide amino lipids and amphiphilic zwitterionic amino lipids
#1842COMPOSITIONS AND METHODS FOR GENE EDITING FOR HEMOPHILIA A
#1843COMPOSITIONS AND METHODS FOR FIBROBLAST GROWTH FACTOR RECEPTOR 3-MEDIATED DELIVERY TO ASTROCYTES
#1844Extracellular Vesicles From Human Induced Pluroptent Stem Cells
#1845MICELLAR NANOPARTICLES AND USES THEREOF
#1846GENETICALLY ENGINEERED SWINE FOR PRECLINICAL VALIDATION
#1847SYSTEMS AND METHODS FOR TARGETED INTEGRATION AND GENOME EDITING AND DETECTION THEREOF USING INTEGRATED PRIMING SITES
#1848RNA-GUIDED NUCLEIC ACID MODIFYING ENZYMES AND METHODS OF USE THEREOF
#1849COMPOSITIONS AND METHODS FOR RNA-ENCODED DNA-REPLACEMENT OF ALLELES
#1850COMPOSITIONS AND METHODS FOR ENHANCING BIOMASS PRODUCTIVITY IN PLANTS
#1851CANCER THERAPY
#1852EXTRACELLULAR VESICLE-NLRP3 ANTAGONIST
#1853RNAi agents for inhibiting expression of complement component C3 (C3), pharmaceutical compositions thereof, and methods of use
#1854METHODS AND COMPOSITIONS FOR REJUVENATING CNS GLIAL POPULATIONS BY SUPPRESION OF TRANSCRIPTION FACTORS
#1855METHOD OF PRODUCING HAIRPIN SINGLE-STRANDED RNA MOLECULE
#1856Methods for Treatment of Alport Syndrome
#1857NUCLEIC ACID DELIVERY TO THE CENTRAL NERVOUS SYSTEM
#1858METHODS AND COMPOSITIONS FOR ACCELERATING OLIGODENDROCYTE MATURATION
#1859MODIFIED GUIDE RNAS FOR CRISPR GENOME EDITING
#1860METHODS OF TREATING OSMIDROSIS
#1861COMPOSITIONS AND METHODS OF NUCLEIC ACID-TARGETING NUCLEIC ACIDS
#1862CASZ COMPOSITIONS AND METHODS OF USE
#1863COMPOSITIONS AND METHODS FOR INHIBITION OF CELL-PENETRATING ANTIBODIES
#1864PHARMACEUTICAL USE OF FAM19A5 INVOLVED IN REGULATING GLIOGENESIS
#1865Transcriptome In Vivo Analysis (TIVA) and Transcriptome In Situ Analysis (TISA)
#1866Sequence specific antimicrobials
#1867Conjugated Antisense Compounds for Use in Therapy
#1868LIPID NANOPARTICLE PREPARATION METHOD AND PREPARATION APPARATUS THEREFOR
#1869OLIGONUCLEIC ACID VARIANT LIBRARIES AND SYNTHESIS THEREOF
#1870SYSTEMS AND METHODS FOR DETERMINING BARCODES AND SCREENING IN SITU
#1871COMPOSITIONS AND METHODS FOR RNA-ENCODED DNA-REPLACEMENT OF ALLELES
#1872REPRESSOR PROTEINS FOR GENE REGULATION AND CRISPR INTERFERENCE
#1873Composition Comprising Antisense Oligonucleotide and Use Thereof for Treatment of Duchenne Muscular Dystrophy
#1874METHOD OF TREATING FATTY LIVER DISEASE
#1875CHIMERIC DOUBLE-STRANDED NUCLEIC ACID
#1876NUCLEIC ACIDS SIMULTANEOUSLY INHIBITING EXPRESSION OF C-MET GENE AND PD-L1 GENE
#1877METHODS AND COMPOSITIONS USED TO MODIFY CHROMATIN ARCHITECTURE TO REGULATE PHENOTYPE IN AGING AND CANCER
#1878USE OF miRNA408 IN REGULATION OF CADMIUM ACCUMULATION IN CROP
#1879ANTI-TRANSFERRIN RECEPTOR ANTIBODIES AND USES THEREOF
#1880METHODS OF RESTORING FUNCTIONAL CAPACITY AND LINEAGE COMPOSITION OF AN AGING BLOOD AND VASCULAR SYSTEM
#1881PLASMONICS SENSING NANOPLATFORMS FOR HUMAN STEM CELL APPLICATIONS AND METHODS THEREOF
#1882Methods and Compositions for Modifying a Mutant Dystrophin Gene in a Cell's Genome
#1883SYNTHETIC NUCLEIC ACIDS INCLUDING ASTROCYTE-DIRECTED PROMOTER CONSTRUCTS AND METHODS OF USING THE SAME
#1884WPRE mutant constructs, compositions, and methods thereof
#1885MULTI-CONJUGATE OF SIRNA AND PREPARING METHOD THEREOF
#1886METHODS FOR MULTIPLEXING RECOMBINASE POLYMERASE AMPLIFICATION
#1887Modified Guide RNAs Comprising an Internal Linker for Gene Editing
#1888ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#1889Splicing Modulators for the Treatment of Timothy Syndrome
#1890USE OF FUBP1 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#1891ANTISENSE OLIGONUCLEOTIDES TARGETING FOXG1
#1892OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#1893MODULATING REGULATORY T CELL FUNCTION IN AUTOIMMUNE DISEASE AND CANCER
#1894GUIDE RNA FOR EDITING POLYADENYLATION SIGNAL SEQUENCE OF TARGET RNA
#1895OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME
#1896VECTOR SYSTEMS AND METHODS OF USING SAME
#1897OLIGONUCLEOTIDE FOR INDUCING N-EXON SKIPPING DURING REST MRNA PRECURSOR PROCESSING
#1898PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1899Compositions and methods for organ specific delivery of nucleic acids
#1900COMPOSITIONS AND METHODS FOR TREATING CEP290 ASSOCIATED DISEASE
#1901VIRAL VECTOR-BASED RNA DELIVERY SYSTEM AND USE THEREOF
#1902MODULATION OF GYS1 EXPRESSION
#1903ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE
#1904METHODS FOR TREATMENT OF POLYCYSTIC KIDNEY DISEASE
#1905USING siRNAs AGAINST TAU CIRCULAR RNAS AS A RATIONAL THERAPY FOR ALZHEIMER'S DISEASE
#1906ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT
#1907RNA DELIVERY SYSTEM FOR TREATMENT OF HUNTINGTON'S DISEASE
#1908TARGETED INHIBITION USING ENGINEERED OLIGONUCLEOTIDES
#1909CD70-TARGETED MICELLES ENHANCE HIF2? siRNA DELIVERY AND INHIBIT ONCOGENIC FUNCTIONS IN PATIENT-DERIVED CLEAR CELL RENAL CARCINOMA CELLS
#1910RNA PLASMID DELIVERY SYSTEM AND APPLICATION THEREOF
#1911Selective Antisense Compounds and Uses Thereof
#1912RNA INTERFERENCE DELIVERY FORMULATION AND METHODS FOR MALIGNANT TUMORS
#1913SYSTEMS AND METHODS FOR GENOME-WIDE ANNOTATION OF GENE REGULATORY ELEMENTS LINKED TO CELL FITNESS
#1914ANTISENSE OLIGONUCLEOTIDES FOR USE IN THE TREATMENT OF CORNEAL DYSTROPHIES
#1915Oligonucleotide Comprising Inosine for Treating DMD
#1916RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE
#1917TARGETED RNA EDITING
#1918COMPOSITIONS, METHODS, MODULES AND INSTRUMENTS FOR AUTOMATED NUCLEIC ACID-GUIDED NUCLEASE EDITING IN MAMMALIAN CELLS VIA VIRAL DELIVERY
#1919GENERATION OF NOVEL CRISPR GENOME EDITING AGENTS USING COMBINATORIAL CHEMISTRY
#1920HSD17B13 VARIANTS AND USES THEREOF
#1921MESENCHYMAL STEM CELL HAVING OXIDATIVE STRESS RESISTANCE, PREPARATION METHOD THEREFOR, AND USE THEREOF
#1922METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS
#1923TREATMENT AND DIAGNOSIS OF IMMUNE DISORDERS
#1924COMPOSITIONS AND METHODS FOR RECOMBINANT PARVOVIRUS PRODUCTION
#1925MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF NERVOUS SYSTEM DYSFUNCTION
#1926NUCLEIC ACID MOLECULES FOR PSEUDOURIDYLATION
#1927COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#1928MODIFIED OLIGONUCLEOTIDES TARGETING SNPs
#1929PROTEIN ARGININE METHYLTRANSFERASE 9 INHIBITORS AND METHODS OF USE
#1930COMPLEMENT COMPONENT 9 (C9) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1931MODULATION OF TRANSTHYRETIN EXPRESSION
#1932ADENOSINE DEAMINASE BASE EDITORS AND METHODS OF USING SAME TO MODIFY A NUCLEOBASE IN A TARGET SEQUENCE
#1933Synergistic Genome-Nonintegrating Reprogramming by Micrornas and Transcription Factors
#1934Compositions and methods for improved malonyl-CoA biosynthesis using 2-stage dynamic metabolic control
#1935Compositions and methods of treating facioscapulohumeral muscular dystrophy
#1936TARGETED DNA DEMETHYLATION AND METHYLATION
#1937METHOD OF TREATMENT OF MALARIA BY TARGETTING OPEN READING FRAMES
#1938Methods and products for genetic engineering
#1939PEPTIDIC BLOCKS FOR NUCLEIC ACID DELIVERY
#1940CATIONIC AMPHIPHILIC POLYMERS FOR CODELIVERY OF HYDROPHOBIC AGENTS AND NUCLEIC ACIDS
#1941COMPOSITIONS AND METHODS FOR TARGETED RNA DELIVERY
#1942COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#1943MIR200C-EPCAM AXIS REPROGRAMED IMMUNE CELLS FOR ENHANCED ANTI-TUMOR FUNCTION
#1944USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#1945INHIBITION OF EXPANSION AND FUNCTION OF PATHOGENIC AGE-ASSOCIATED B CELLS AND USE FOR THE PREVENTION AND TREATMENT OF AUTOIMMUNE DISEASE
#1946MICELLAR NANOPARTICLES AND USES THEREOF
#1947NUCLEASE-MEDIATED GENOME EDITING OF PRIMARY CELLS AND RELATED KITS
#1948COMPOSITIONS FOR AND METHODS OF ENGINEERING THE TRANSCRIPTOME
#1949RNA CLEAVAGE-INDUCED TRANSCRIPT STABILIZER AND USES THEREOF
#1950COMPOUNDS FOR TREATMENT OF OSTEOARTHRITIS
#1951RNAI CONJUGATES AND USES THEREOF
#1952C/EBP Alpha Short Activating RNA Compositions and Methods of Use
#1953COMPOSITIONS AND METHODS FOR IMPROVED GENE EDITING
#1954GENETICALLY MODIFIED CELLS AND USES THEREOF FOR PREVENTION OF ACUTE GRAFT-VERSUS-HOST DISEASE
#1955Compositions and methods of treating facioscapulohumeral muscular dystrophy
#1956COMPOSITIONS AND METHODS FOR THE TARGETING OF PCSK9
#1957COMPOSITIONS AND METHODS FOR THE TARGETING OF PCSK9
#1958METHODS AND KITS FOR DETECTING A RISK FOR DEVELOPING NEUROLOGICAL OR NEUROPHYSIOLOGICAL DISORDERS
#1959METHODS FOR GENETIC CONTROL OF INSECT INFESTATIONS IN PLANTS AND COMPOSITIONS THEREOF
#1960METHOD FOR MODULATING PLANT PROCESSES
#1961CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#1962COMPOSITIONS FOR TREATMENT OF CONDITIONS AND DISEASES ASSOCIATED WITH POLYCYSTIN EXPRESSION
#1963EXPRESSION OF FOXP3 IN EDITED CD34+ CELLS
#1964COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
#1965USE OF MIRNA-485 INHIBITOR TO REGULATE PSD95, SYNAPTOPHYSIN, AND CASPASE-3 EXPRESSION
#1966iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)
#1967COAGULATION FACTOR X (F10) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1968OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#1969MODIFIED HETERO NUCLEIC ACIDS
#1970METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF A SUBJECT IN NEED THEREOF
#1971COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY
#1972MODIFIED OLIGONUCLEOTIDES
#1973COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#1974ENHANCED CHIMERIC ANTIGEN RECEPTOR FOR IMMUNE EFFECTOR CELL ENGINEERING AND USE THEREOF
#1975Methods for Treatment of Alport Syndrome
#1976LIVER-SPECIFIC DRUG DELIVERY CARRIER COMPRISING NUCLEIC ACID NANOPARTICLE AND CHOLESTEROL AND USE THEREOF
#1977TARGETING CHROMOSOMAL INSTABILITY AND DOWNSTREAM CYTOSOLIC DNA SIGNALING FOR CANCER TREATMENT
#1978Advanced Cell-Permeable Peptide Carriers
#1979METHOD OF PRODUCING HAIRPIN SINGLE-STRANDED RNA MOLECULES
#1980INDUCIBLE ANTI-SENSE REPRESSOR SWITCHES AND USES THEREOF
#1981MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#1982ANTIFIBROTIC AND ANTITUMOR ACTIVITY OF CD63 BLOCKADE
#1983GENOMIC EDITING OF COMPLEMENT
#1984SUBSTANCES AND METHODS FOR TREATING DYSTROPHIC EPIDERMOLYSIS BULLOSA
#1985COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES
#1986SYSTEMS AND METHODS FOR TREATING ALPHA 1-ANTITRYPSIN (A1AT) DEFICIENCY
#1987ENZYMES WITH RUVC DOMAINS
#1988Methods and products for genetic engineering
#1989OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1990ENGINEERED EXTRACELLULAR VESICLES AND THEIR USES
#1991COMBINATION siRNA AND PEPTIDE DOCKING VEHICLE (PDoV) COMPOSITIONS AND METHODS OF THEIR USE FOR IMPROVED REGULATION AND FUNCTIONALITY
#1992METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY
#1993PNMA2-BASED CAPSIDS AND USES THEREOF
#1994Microbiome modulation of a host by delivery of DNA payloads with minimized spread
#1995Tuning cascade assay kinetics via molecular design
#1996Treatment Of Ophthalmic Conditions With Son of Sevenless 2 (SOS2) Inhibitors
#1997Compounds and methods for modulating SCN2A
#1998OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#1999Novel Structurally Designed shRNAs
#2000ISOLATED DOUBLE STRANDED DNA POLYNUCLEOTIDE
#2001CONJUGATED OLIGONUCLEOTIDE COMPOUNDS, METHODS OF MAKING AND USES THEREOF
#2002REGULATORY SYSTEM FOR EXPRESSION OF A GENE OF INTEREST IN A TARGET CELL AND METHOD OF USE THEREOF
#2003GENE THERAPY FOR AADC DEFICIENCY
#2004COMPOSITIONS AND METHODS FOR THE TARGETING OF PTBP1
#2005Compositions and methods for targeted RNA delivery
#2006MODULATION OF AAV-BASED GENE EXPRESSION
#2007ISOLATED RECOMBINANT ONCOLYTIC ADENOVIRUSES, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF FOR DRUGS FOR TREATMENT OF TUMORS AND/OR CANCERS
#2008COMPOSITIONS AND METHODS FOR TREATING AGE-RELATED MACULAR DEGENERATION AND GEOGRAPHIC ATROPHY
#2009METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS
#2010ARTIFICIALLY SYNTHESIZED SPHINGOSINE DERIVATIVE LIPOID MONOMER AND USE OF SAME FOR DELIVERING NUCLEIC ACID
#2011EUKARYOTIC CELLS FOR PROTEIN MANUFACTURING AND METHODS OF MAKING THEM
#2012NANOPARTICLE COMPOSITIONS CONTAINING SUGAR FUNCTIONALIZED NUCLEIC ACID CARRIERS
#2013ULTRAPURE MINIVECTORS FOR GENE THERAPY
#2014COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#2015MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#2016NUCLEIC ACID MOLECULES AND THEIR METHODS OF USE
#2017MIR-7-5P MIMIC FOR INHIBITING MIGRATION AND INVASION OF BREAST CANCER, SCREENING METHOD AND APPLICATION THEREOF
#2018DEAD GUIDES FOR CRISPR TRANSCRIPTION FACTORS
#2019ANTISENSE OLIGONUCLEOTIDES INCREASING FOXG1 EXPRESSION
#2020COMPOSITIONS AND METHODS FOR TREATING DISEASE ASSOCIATED WITH DUX4 OVEREXPRESSION
#2021ENGINEERED NUCLEIC ACIDS TARGETING LONG NONCODING RNA INVOLVED IN PATHOGENIC INFECTION
#2022VECTORS COMPRISING STUFFER POLYNUCLEOTIDE SEQUENCES
#2023RNAi AGENT TARGETING MYD88 AND USE THEREOF
#2024METHODS OF MEAT PRODUCTION BY IN VITRO CELL CULTIVATION
#2025MODIFIED T CELLS FOR ADOPTIVE IMMUNOTHERAPY
#2026METHOD OF MODULATING CELL PROLIFERATION
#2027COMPOSITIONS AND METHODS FOR UPREGULATING ISOFORMS OF DYSTROPHIN AS THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY (DMD)
#2028Compositions and methods of treating ocular diseases
#2029Heterocyclic carboxylate compounds as glycolate oxidase inhibitors
#2030OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#2031Crispr enzymes and systems
#2032RIBOSOMAL RNA SCAFFOLDS FOR PROTEIN-FREE AND TEMPLATE-FREE SYNTHESIS OF PEPTIDES
#2033Methods and Systems for Guide RNA Design and Use
#2034ANTISENSE OLIGOMERS TARGETING PCSK9
#2035LOCALIZED THERAPY OF LOWER AIRWAYS INFLAMMATORY DISORDERS WITH PROINFLAMMATORY CYTOKINE INHIBITORS
#2036COMPOSITION AND METHOD FOR INHIBITING ANGIOTENSINOGEN (AGT) PROTEIN EXPRESSION
#2037AAV TREATMENT OF HUNTINGTON’S DISEASE
#2038RNAi TARGETING OF FUNGAL PATHOGEN TETRASPANIN PROTEINS
#2039RNAI CONSTRUCTS AND METHODS FOR INHIBITING FAM13A EXPRESSION
#2040MIRNA COMPOSITION COMPRISING 11 SPECIFIC MIRNAS AND ITS USE IN THE TREATMENT OF CANCER
#2041DRUG DELIVERY COMPOSITION, METHOD FOR PRODUCING SAME AND USE THEREOF
#2042Treatment Of Endometriosis With R-Spondin 3 (RSPO3) Inhibitors
#2043CONJUGATED OLIGONUCLEOTIDES
#2044SINGLE-STRANDED OLIGONUCLEOTIDE
#2045CRISPR/Cas screening platform to identify genetic modifiers of tau seeding or aggregation
#2046METHOD OF ASSESSING ACTIVITY OF RECOMBINANT ANTIGEN RECEPTORS
#2047GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#2048GENETIC THERAPY FOR GLAUCOMA AND OPTIC NEUROPATHIES
#2049COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION
#2050Altering microbial populations and modifying microbiota
#2051TOXIC RNAi ACTIVE SEED SEQUENCES FOR KILLING CANCER CELLS
#2052ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#2053cGMP exosome loaded therapeutics for treating sickle cell disease
#2054RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING AMYOTROPHIC LATERAL SCLEROSIS
#2055APPLICATION OF ANTISENSE OLIGONUCLEOTIDE TARGETING PBX1 PROMOTER REGION G-QUADRUPLEX IN PREPARATION OF MEDICINE FOR TREATING MELANOMA
#2056Immunomodulators Targeting MORC3 for Interferon Induction
#2057REGULATORY ELEMENTS FOR SCHWANN CELL-SPECIFIC GENE EXPRESSION
#2058FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2059PEPTIDE-NUCLEIC ACID COMPLEX HAVING BLOOD-BRAIN BARRIER PENETRATION ABILITY AND COMPOSITION COMPRISING SAME
#2060Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#2061VARIANTS OF CAS12A NUCLEASES AND METHODS OF MAKING AND USE THEREOF
#2062VARIANTS OF CAS12A NUCLEASES AND METHODS OF MAKING AND USE THEREOF
#2063Models of tauopathy
#2064METHODS AND COMPOSITIONS FOR TREATING TUMOR CELLS
#2065IN UTERO CRISPR-MEDIATED THERAPEUTIC EDITING OF GENES
#2066ROR2 INHIBITORS AND USE THEREOF IN TREATING AND/OR PREVENTING CARTILAGE LOSS
#2067COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS
#2068TRANS-SPLICING RNA (tsRNA)
#2069TRIPLE FUNCTION ADENO-ASSOCIATED VIRUS (AAV)VECTORS FOR THE TREATMENT OF C9ORF72 ASSOCIATED DISEASES
#2070OPTIMIZED ANTI-FLT1 OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS
#2071GATA6-AS1 lncRNA FOR USE IN THERAPY
#2072ORAL DELIVERY OF ANTISENSE CONJUGATES TARGETING PCSK9
#2073METHODS AND COMPOSITIONS FOR MODULATING APOLIPOPROTEIN (A) EXPRESSION
#2074COMPOSITIONS AND METHODS FOR TREATMENT OF CARDIAC DISEASES
#2075Compounds and methods for modulating ATXN1
#2076Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#2077Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
#2078Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide
#2079ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS WITH IMPROVED RETINAL TRANSDUCTION AND USES THEREOF
#2080Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
#2081Muscle targeting complexes and uses thereof for treating dystrophinopathies
#2082NOVEL FATTY ACIDS AND THEIR USE IN CONJUGATION TO BIOMOLECULES
#2083Lipid compositions
#2084PROTOPARVOVIRUS AND TETRAPARVOVIRUS COMPOSITIONS AND METHODS FOR GENE THERAPY
#2085METHODS AND COMPOSITIONS FOR GENE EDITING IN HEMATOPOIETIC STEM CELLS
#2086METHODS AND COMPOSITIONS FOR CONTROLLING MERISTEM SIZE FOR CROP IMPROVEMENT
#2087POLY-MORPHOLINO OLIGONUCLEOTIDE GAPMERS
#2088Method for Producing Naive Human IPS Cells From Somatic Cells
#2089TRANSFERRIN RECEPTOR BINDING PROTEINS AND CONJUGATES
#2090ANTISENSE COMPOUNDS
#2091APTAMER-siRNA FUSIONS
#2092COMPOSITIONS AND METHODS TO TREAT CANCER
#2093DOUBLE STRANDED RNA TARGETING ANGIOTENSINOGEN (AGT) AND METHODS OF USE THEREOF
#2094COMPLEX FOR TREATING OPTIC NERVE DISEASE, AND PREPARATION METHOD THEREFOR AND USE THEREOF
#2095METHODS FOR PRODUCING EXTRACELLULAR VESICLES ENRICHED IN ANTI-INFLAMMATORY MICRORNAS
#2096PHARMACEUTICAL COMPOSITION
#2097OLIGONUCLEOTIDES FOR PMS1 MODULATION
#2098CARDIOMYOCYTE-DERIVED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USE THEREOF
#2099IN VIVO METHODS FOR SELECTING PEPTIDES THAT CROSS THE BLOOD BRAIN BARRIER, RELATED COMPOSITIONS AND METHODS OF USE
#2100LIPID NANOPARTICLE