109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
SYSTEMS AND METHODS FOR IDENTIFYING CELLS THAT HAVE UNDERGONE GENOME EDITING
#2402GENE THERAPIES FOR LYSOSOMAL DISORDERS
#2403MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR OVARIAN CANCER
#2404METHOD FOR ACTIVATING EXPRESSION OF GAMMA-GLOBIN GENE, AND COMPOSITION
#2405TARGETED REPLACEMENT OF ENDOGENOUS T CELL RECEPTORS
#2406HIGH-EFFICIENCY SCREENING METHOD FOR RNA-TARGETING DRUGS USING NANOPORES
#2407COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION
#2408VECTORS AND METHODS FOR IN VIVO TRANSDUCTION
#2409Modified oligonucleotides
#2410COMPOSITIONS AND METHODS OF TREATMENT OF MUSCLE DISORDERS BY TARGETING H19X-ENCODED NON-CODING RNAS
#2411ANTI-SEED PNAS AND MICRORNA INHIBITION
#2412Micro-Vesicles Comprising Cargo Prodrug RNA and Methods of Using the Same
#2413EXPRESSION CONTROL USING A REGULATABLE INTRON
#2414TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#2415IN VITRO GENETIC DISEASE MODEL CELL AND METHOD FOR PRODUCING THE SAME
#2416COMPOSITIONS AND METHODS FOR ENHANCING NUCLEIC ACID THERAPEUTICS
#2417ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN STRIATAL NEURONS
#2418High sterol-containing lipid nanoparticles
#2419Compositions and methods for targeted delivery to cells
#2420RNAS for complement inhibition
#2421Blockade of miR466l-3p binding to IL-17A mRNA with site-specific target site blocker prevents neuro-inflammatory-mediated disease
#2422COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
#2423REPEAT RNA AS BIOMARKERS OF TUMOR IMMUNE RESPONSE
#2424METHODS AND COMPOSITIONS FOR THE TREATMENT OF RETINOPATHY AND OTHER OCULAR DISEASES
#2425LOADING OF EXTRACELLULAR VESICLES THROUGH IMPARTING OF MECHANICAL SHEAR
#2426NUTRITIONAL COMPOSITION COMPRISING MIR-3141
#2427Compositions and methods for mitigating pest infestation
#2428Oligonucleotides for inducing paternal UBE3A expression
#2429COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#2430TARGETING PEPTIDES FOR DIRECTING ADENO-ASSOCIATED VIRUSES (AAVs)
#2431Artificial genome manipulation for gene expression regulation
#2432CURING FOR RECURSIVE NUCLEIC ACID-GUIDED CELL EDITING
#2433METHODS OF CONTROLLING RED BLOOD CELL PRODUCTION
#2434MICRORNAS AND METHODS OF THEIR USE
#2435GalNAc compositions for improving siRNA bioavailability
#2436ANTI-C9ORF72 OLIGONUCLEOTIDES AND RELATED METHODS
#2437NUCLEIC ACID COMPLEX
#2438Novel Replicase Cycling Reaction (RCR) and the Related SamRNA Designs Thereof
#2439Targeted inhibition using engineered oligonucleotides
#2440MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#2441RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE
#2442COMPOSITIONS AND METHODS FOR SILENCING MYOC EXPRESSION
#2443OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#2444Pseudotyped viral particles, compositions comprising the same, and uses thereof
#2445IONIZABLE CATIONIC LIPIDS FOR RNA DELIVERY
#2446Gene therapy for haploinsufficiency
#2447LIGAND COMPOUNDS, CONJUGATES, AND APPLICATIONS THEREOF
#2448MICRORNA AND USES THEREOF IN PREVENTION AND/OR TREATMENT OF FIBROPLASIA MEDICAL SIGN AND/OR SYNDROME
#2449COMPOSITIONS AND METHODS TO CONTROL INSECT PESTS
#2450METHODS FOR DIAGNOSING HUNTINGTON’S DISEASE
#2451SEQUENTIAL GENE EDITING IN PRIMARY IMMUNE CELLS
#2452COMPOSITIONS AND METHODS FOR HEMOGLOBIN PRODUCTION
#2453Tuning cascade assay kinetics via molecular design
#2454Triggering Receptor Expressed On Myeloid Cells 2 (TREM2) Variants And Uses Thereof
#2455MAGNETIC INORGANIC IRON-BASED NANOPARTICLES
#2456Compositions and methods of treating facioscapulohumeral muscular dystrophy
#2457DUCHENNE MUSCULAR DYSTROPHY-RELATED EXONIC SPLICING ENHANCER, sgRNA AND GENE EDITING TOOL, AND APPLICATIONS
#2458MODIFIED SIRNA WITH REDUCED OFF-TARGET ACTIVITY
#2459MUCOPENETRATING FORMULATIONS
#2460COMBINATORY TREATMENT OF SMA WITH SARNA AND MRNA MODULATORS
#2461COMBINED THERAPY AGAINST CANCER
#2462TARGETED DELIVERY OF AN INHIBITOR OF MIR-21 TO MACROPHAGES FOR THE TREATMENT OF PULMONARY FIBROSIS
#2463Oligonucleotide Agonists Targeting Progranulin
#2464METHODS FOR ENGINEERING NON-NEURONAL CELLS INTO NEURONS AND USING NEWLY ENGINEERED NEURONS TO TREAT NEURODEGENERATIVE DISEASES
#2465OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#2466COMPOSITIONS AND METHODS FOR TREATING NEURODEGENERATIVE DISEASES
#2467NUCLEIC ACID CONSTRUCTS FOR DELIVERING POLYNUCLEOTIDES INTO EXOSOMES
#2468MULTIMERIC OLIGONUCLEOTIDES WITH ENHANCED BIOACTIVITY
#2469CRISPR/CAS FUSION PROTEINS AND SYSTEMS
#2470PHARMACEUTICAL COMPOSITIONS FOR TREATMENT OF MICRORNA RELATED DISEASES
#2471Gene editing for hemophilia A with improved factor VIII expression
#2472Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
#2473Treatment delivery system and method
#2474METHODS FOR TREATING TRIPLE-NEGATIVE BREAST CANCER
#2475COMPOSITIONS AND METHODS FOR TRANSDIFFERENTIATING CELLS
#2476CDC20 VARIANTS RESISTANT TO ANTI-MITOTIC DRUGS AND RELATED METHODS AND COMPOSITIONS
#2477METHOD FOR THE PRODUCTION OF DOUBLE-STRANDED RNA
#2478GENOMIC SAFE HARBORS FOR GENETIC THERAPIES IN HUMAN STEM CELLS AND ENGINEERED NANOPARTICLES TO PROVIDE TARGETED GENETIC THERAPIES
#2479COMPOSITIONS COMPRISING CURONS AND USES THEREOF
#2480MODIFYING THE SPECIFICITY OF PLANT NON-CODING RNA MOLECULES FOR SILENCING GENE EXPRESSION
#2481COMPOSITIONS AND METHODS COMPRISING ENGINEERED SHORT NUCLEAR RNA (SNRNA)
#2482Oligomeric Compounds Comprising Bicyclic Nucleotides and Uses Thereof
#2483Compositions and methods of treating Facioscapulohumeral muscular dystrophy
#2484COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#2485Treatment of Airway Conditions by Modulation of MiR200 Family MicroRNAs
#2486Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#2487Pseudotyped viral particles, compositions comprising the same, and uses thereof
#2488Genetically-modified immune cells comprising a microRNA-adapted shRNA (shRNAmiR)
#2489MOTOR NEURON-SPECIFIC EXPRESSION VECTORS
#2490DETECTION ASSAYS
#2491GENOMIC EDITING WITH SITE-SPECIFIC RETROTRANSPOSONS
#2492METHODS AND COMPOSITIONS FOR EVOLVING BASE EDITORS USING PHAGE-ASSISTED CONTINUOUS EVOLUTION (PACE)
#24933'-UTR SEQUENCES FOR STABILIZATION OF RNA
#2494Polypeptides useful for gene editing and methods of use
#2495METHODS FOR IMPROVING THE HEALTH OF PORCINE SPECIES BY TARGETED INACTIVATION OF CD163
#2496ENGINEERED MICROALGAE FEED TO IMPROVE HONEY BEE PATHOGEN RESISTANCE AND NUTRITION
#2497RNA-DIRECTED DNA CLEAVAGE BY THE Cas9-crRNA COMPLEX
#2498Compositions and methods for modulating APOC3 expression
#2499METHODS OF TFEB ACTIVATION AND LYSOSOMAL BIOGENESIS AND COMPOSITIONS THEREFOR
#2500COMPOSITIONS AND METHODS FOR HEMOGLOBIN PRODUCTION
#2501CIRCULAR miRNA SPONGES
#2502MIR-96-5P INHIBITOR AND PHARMACEUTICAL COMPOSITION CONTAINING SAME
#2503COMPOSITIONS AND METHODS FOR TREATING DISORDERS ASSOCIATED WITH LOSS-OF-FUNCTION MUTATIONS IN SCN2A
#2504AGENT FOR PREVENTING OR TREATING MUSCULAR DISEASE
#2505siRNAs WITH VINYLPHOSPHONATE AT THE 5' END OF THE ANTISENSE STRAND
#2506METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF RETINOCHISIN 1 (RS1)
#2507METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF GAP JUNCTION PROTEIN BETA 2 (GJB2)
#2508COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING COMPLEMENT COMPONENT C3-ASSOCIATED DISEASES
#2509SINGLE-STRANDED POLYNUCLEOTIDE
#2510Engineered Guide RNA Sequences for In Situ Detection and Sequencing
#2511Methods and Compositions for the Single Tube Preparation of Sequencing Libraries Using Cas9
#2512MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#2513Solid support for synthesizing nucleic acid sequences and methods for making and using
#2514Muscle targeting complexes and uses thereof for treating dystrophinopathies
#2515CD133 RELATED TO ANTICANCER AGENT RESISTANCE IN COLON CANCER AND USE THEREOF
#2516RNA Replicon for Versatile and Efficient Gene Expression
#2517COMBINATORIAL INHIBITION OF TRANSCRIPTION FACTORS FOR TREATMENT OF HEART FAILURE
#2518OLIGONUCLEOTIDES, MANUFACTURING METHOD FOR SAME, AND TARGET RNA SITE-SPECIFIC EDITING METHOD
#2519RNAi agents for inhibiting expression of DUX4, compositions thereof, and methods of use
#2520SKELETAL MUSCLE DELIVERY PLATFORMS AND METHODS OF USE THEREOF
#2521Modulators of APOL1 expression
#2522Treatment of Genetic Dilated Cardiomyopathies
#2523COMBINATORIAL INHIBITION OF MIRNAS FOR TREATMENT OF HEART FAILURE
#2524lncRNA-REGULATED GENE EXPRESSION SYSTEM
#2525METHODS OF TREATING AND PREVENTING BACTERIAL INFECTIONS
#2526EFFICIENT RNA SWITCHES AND RELATED EXPRESSION SYSTEMS
#2527ISOLATED RECOMBINANT ONCOLYTIC POXVIRUS CAPABLE OF BEING REGULATED AND CONTROLLED BY MICRORNA AND USE THEREOF
#2528COMPOSITIONS AND METHODS FOR TREATING AND PREVENTING INFLAMMATION
#2529METHODS AND COMPOSITIONS FOR TREATING AND/OR PREVENTING A DISEASE OR DISORDER ASSOCIATED WITH ABNORMAL LEVEL AND/OR ACTIVITY OF THE IFP35 FAMILY OF PROTEINS
#2530NUCLEOSIDE DERIVATIVE AND USE THEREOF
#2531Antiviral Agent
#2532Genetically engineered T cells with Regnase-1 and/or TGFBRII disruption have improved functionality and persistence
#2533Orthogonal Cas9 Proteins for RNA-Guided Gene Regulation and Editing
#2534METHODS AND COMPOSITIONS FOR TRANSDUCING LYMPHOCYTES AND REGULATING THE ACTIVITY THEREOF
#2535AAV DELIVERY SYSTEM FOR LUNG CANCER TREATMENT
#2536Promoter of Hspa5 Gene
#2537Complement factor B (CFB) iRNA compositions and methods of use thereof
#2538USE OF A1CF INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#2539Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#2540TARGETING ZNF410 FOR FETAL HEMOGLOBIN INDUCTION IN BETAHEMOGLOBINOPATHIES
#2541Circular siRNAs
#2542TRUNCATED PROMOTOR FOR RECOMBINANT GENE EXPRESSION
#2543USE OF P38 INHIBITORS TO REDUCE EXPRESSION OF DUX4
#2544RNA-guided nucleases and active fragments and variants thereof and methods of use
#2545Method for Retaining Splicing RNAs in the Nucleus Based on Chemically Modified Antisense Oligonucleotides
#2546Compositions and methods for inhibiting expression of transthyretin
#2547Cationic lipids
#2548COMPOSITIONS AND METHODS FOR PREPARING AN ALZHEIMER'S DISEASE ANIMAL MODEL USING MICRORNA
#2549METHODS AND COMPOSITIONS FOR THE TREATMENT OF MUSCULAR DYSTROPHY
#2550MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT
#2551Nucleic acid oligomers and uses therefor
#2552Use of Paperclip RNA Structure to Inhibit Target Gene Expression
#2553DIAGNOSIS AND TREATMENT OF CHRONIC DIABETIC COMPLICATIONS USING LONG NONCODING RNAS AS TARGETS
#2554RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE
#2555OPA1 antisense oligomers for treatment of conditions and diseases
#2556Method and composition for early detection of malignancies
#2557NUTRITIONAL COMPOSITION COMPRISING MIR-3126
#2558METHOD FOR TREATING AND PROGNOSING CANCER LIKE GLIOBLASTOMA
#2559Use of PIWI-interacting RNA piR-hsa-211106
#2560Composition for regulating expression of PROX1 or expression of telomerase reverse transcriptase comprising activity regulator or method for screening telomerase reverse transcriptase regulator
#2561GENOME EDITING OF HUMAN NEURAL STEM CELLS USING NUCLEASES
#2562COMPOSITIONS, METHODS, MODULES AND INSTRUMENTS FOR AUTOMATED NUCLEIC ACID-GUIDED NUCLEASE EDITING IN MAMMALIAN CELLS USING MICROCARRIERS
#2563METHOD FOR SELECTING CELL
#2564COMPOSITIONS AND METHODS FOR THE TREATMENT OF CANCER
#2565NUTRITIONAL COMPOSITION COMPRISING MIR-3184
#2566SYNTHETIC RNA FRAGMENT AND ITS USES FOR RNA-DEPENDENT AMPLIFICATION
#2567METHODS AND HYBRIDS FOR TARGETED NUCLEIC ACID EDITING IN PLANTS USING CRISPR/CAS SYSTEMS
#2568STING-DEPENDENT ACTIVATORS FOR TREATMENT OF DISEASE
#2569METHODS AND COMPOSITIONS RELATED TO CATALYTIC ACTIVATION OF HUMAN ARGONAUTE-3
#2570MicroRNA-TARGETED THERAPY FOR CARDIAC REPAIR
#2571METHODS AND COMPOSITIONS RELATING TO ENGINEERED GUIDE SYSTEMS FOR ADENOSINE DEAMINASE ACTING ON RNA EDITING
#2572METHODS AND COMPOSITIONS FOR NEUROPROTECTION
#2573COMPOSITION AND METHODS FOR IDENTIFYING ANTISENSE GUIDE RNA FOR RNA EDITING
#2574THYCLOTIDES
#2575Compositions and methods for organ-protective expression and modulation of coding ribonucleic acids
#2576PLURIPOTENT STEM CELL AND DERIVATIVE THEREOF
#2577COMPOSITIONS AND METHODS RELATING TO EXOSOMES DERIVED FROM HUMAN DERMAL PAPILLA CELLS
#2578REJUVENATION TREATMENT OF AGE-RELATED WHITE MATTER LOSS
#2579RNA-guided nucleases and active fragments and variants thereof and methods of use
#2580NUCLEIC ACID-CONTAINING LIPID PARTICLES AND RELATED METHODS
#2581ENHANCEMENT OF THE PRODUCTION OF ADENOIDVIRUS-BASED GENETRANSFER VECTORS
#2582CONTROL OF MEIOTIC CROSSOVER IN MAIZE
#2583Compositions and methods for enhancing biomass productivity in plants
#2584ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDITING WITH ENDOGENOUS ADENOSINE DEAMINASE ACTING ON RNA (ADAR)
#2585NOVEL MORPHOLINO OLIGONUCLEOTIDE DERIVATIVES
#2586A DBAIT MOLECULE IN COMBINATION WITH KRAS INHIBITOR FOR THE TREATMENT OF CANCER
#2587METHODS AND PHARMACEUTICAL COMPOSITIONS FOR TREATING OCULAR DISEASES
#2588Compositions and Methods for Treating Huntington's Disease and Related Disorders
#2589NUCLEASE SYSTEMS FOR GENETIC ENGINEERING
#2590Compounds and Methods for Reducing ATXN3 Expression
#2591RNA EDITING INHIBITORS AND METHODS OF USE
#2592ARGONAUTE PROTEIN FROM EUKARYOTES AND APPLICATION THEREOF
#2593NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#2594COMPOSITIONS AND METHODS FOR ENHANCING IMMUNE RESPONSE
#2595MATERIALS AND METHODS FOR TREATMENT OF TITIN-BASED MYOPATHIES AND OTHER TITINOPATHIES
#2596PHARMACEUTICAL COMPOSITION FOR TREATING ALZHEIMER'S DISEASE
#2597Selective inhibition of T follicular helper cells for treatment of autoimmune disorders
#2598COMPOSITIONS FOR INHIBITING 3' REPAIR EXONUCLEASE 2 AND METHODS OF SCREENING FOR SUCH COMPOSITIONS
#2599METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION
#2600Materials and Methods for Treatment of Myotonic Dystrophy Type 1 (DM) and Other Related Disorders
#2601Simultaneous gene editing and haploid induction
#2602METHODS AND COMPOSITIONS FOR TREATING EPILEPSY
#2603COMPOSITION FOR PREVENTING OR TREATING ALZHEIMER'S DISEASE COMPRISING INHIBITOR OF ATLASTIN 2, AND METHOD FOR DIAGNOSING ALZHEIMER'S DISEASE BY DETERMINING ATLASTIN 2
#2604Artificial non-coding RNA module for enhancing nitrogen fixation ability of microorganisms
#2605UNA OLIGOMERS FOR THE TREATMENT OF POLYGLUTAMINE DISEASES
#2606COMPOUND, METHOD AND PHARMACEUTICAL COMPOSITION FOR REGULATING EXPRESSION OF ATAXIN 3
#2607FMRP AND CANCER TREATMENT
#2608COMPOSITIONS AND METHODS FOR ENHANCING ACTIVATION AND CYTOLYTIC ACTIVITY OF CD8+ T CELLS THROUGH DISRUPTION OF THE SAGA (SPT-ADA-GCN5-ACETYLTRANSFERASE) COMPLEX
#2609RNA INTERFERENCE-INDUCING NUCLEIC ACID COMPRISING 8-OXOGUANINE, MODIFIED NUCLEIC ACID BINDING TO MICRORNA COMPRISING 8-OXOGUANINE, AND USES THEREOF
#2610COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#2611Muscle-targeting complex comprising an anti-transferrin receptor antibody linked to an oligonucleotide
#2612METHODS AND COMPOSITIONS FOR MODULATING CELLS AND CELLULAR MEMBRANES
#2613METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS
#2614METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#2615CILP-1 Inhibitors for Use in the Treatment of Dilated Cardiomyopathies
#2616NUCLEIC ACID MOLECULE HAVING IMPROVED STABILITY, AND USE THEREOF
#2617NUCLEIC ACID MOLECULE TARGETING MITF GENE AND USE THEREOF
#2618MULTIMERIC OLIGONUCLEOTIDES WITH DIVIDED STRANDS
#2619D-SERINE TRANSPORT MODIFIER AND SCREENING METHOD THEREOF, AND SCREENING METHOD OF D-SERINE TRANSPORTER PROTEIN
#2620SIRNA CONJUGATE, DOUBLE-STRANDED SIRNA CONJUGATE, SALT THEREOF AND APPLICATION THEREOF
#2621MICRORNA AS A THERAPEUTIC AGENT
#2622OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#2623REGULATION OF GENE EXPRESSION VIA APTAMER-MEDIATED CONTROL OF SELF-CLEAVING RIBOZYMES
#2624GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY
#2625SCALING UP MYOGENIC TISSUE: LATE PASSAGE MYOGENICITY
#2626KIT OR DEVICE AND METHOD FOR DETECTING HIPPOCAMPAL ATROPHY
#2627METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA DIRECTED MODULATION OF TRANSCRIPTION
#2628COMPOSITIONS AND METHODS FOR TREATING HYPERTRIGLYCERIDEMIA
#2629SPLICING-DEPENDENT TRANSCRIPTIONAL GENE SILENCING OR ACTIVATION
#2630MAPT RNA INTERFERENCE AGENTS
#2631Compositions and Methods for Treating Alpha-1 Antitrypsin Deficiency
#2632Construct of self-circularization RNA
#2633Guanosine Analogues for Use in Therapeutics Polynucleotides
#2634COMPOSITIONS AND METHODS FOR DELIVERING POLYNUCLEOTIDES
#2635CELL-PENETRATING PEPTIDE-MICRORNA CONJUGATES FOR INTRACELLULAR CELL DELIVERY
#2636METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF OTOFERLIN (OTOF)
#2637MICRORNA-MEDIATED METHODS FOR REJUVENATING CNS GLIAL POPULATIONS
#2638THERAPEUTICS FOR HAPLOINSUFFICIENCY CONDITIONS
#2639DELIVERY OF GENE EXPRESSION MODULATING AGENTS FOR THERAPY AGAINST CANCER AND VIRAL INFECTION
#2640NUCLEIC ACID MOLECULE FOR TREATING THROMBOCYTOPENIA AND APPLICATION THEREOF
#2641METHODS AND COMPOSITIONS FOR MODULATING ALPHA-1-ANTITRYPSIN EXPRESSION
#2642Methods and Systems of Molecular Recording by Crispr-Cas System
#2643Treatments for retinal disease
#2644NEW USE OF CMTR1 HAVING SIRNA PRODUCTION AND FUNCTION ENHANCING ACTIVITY
#2645NUCLEIC ACID MOLECULES FOR REDUCTION OF PAPD5 OR PAPD7 MRNA FOR TREATING HEPATITIS B INFECTION
#2646CONJUGATE GROUP AND CONJUGATE
#2647RNAi FOR CONTROL OF PHLOEM SAP-FEEDING INSECTS IN CROP PLANTS
#2648TISSUE SELECTIVE TRANSGENE EXPRESSION
#2649SINGLE-STRANDED OLIGONUCLEOTIDE
#2650COMPOSITIONS AND METHODS FOR CONTROLLING LEPTINOTARSA
#2651Modified ribonucleic acids and uses thereof
#2652EXOSOME-DERIVED PIWI-INTERACTING RNA AND METHODS OF USE THEREOF
#2653MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#2654METHODS FOR MODULATING MHC-I EXPRESSION AND IMMUNOTHERAPY USES THEREOF
#2655DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#2656Compositions and Methods Using SNRNA Components
#2657Methods of Rescuing Stop Codons via Genetic Reassignment with ACE-tRNA
#2658EFFECTOR PROTEINS AND METHODS OF USE
#2659MODIFIED ENDONUCLEASES AND RELATED METHODS
#2660Methods of producing muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide
#2661COMPOSITIONS AND METHODS FOR TREATING OCULAR DISORDERS
#2662Compositions and methods of treating muscle atrophy and myotonic dystrophy
#2663Compositions and methods of treating muscle atrophy and myotonic dystrophy
#2664LINKER COMPOUNDS
#2665MODULATORS OF FOXP3 EXPRESSION
#2666METHODS FOR TREATING CANCER BY INHIBITING CARM1
#2667Treatment methods for muscular dystrophy
#2668PEPTIDE NUCLEIC ACID COMPLEX HAVING ENDOSOMAL ESCAPE CAPACITY, AND USE THEREOF
#2669Signal boost cascade assay
#2670Tuning cascade assay kinetics via molecular design
#2671Treatment Of Kidney Diseases With Angiopoietin Like 3 (ANGPTL3) Inhibitors
#2672Application of transgenic stem cell-derived exosome in preparing medicament or whitening cosmetic
#2673OLIGONUCLEOTIDES FOR SPLICE MODULATION OF CARD9
#2674APOLIPOPROTEIN E (APOE) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#2675CARDIAC CELL PROLIFERATION BY ADMINISTERING INHIBITORS OF SAV1, NF2, MOB1 AND/OR MUTANT SRF
#2676Thiomorpholino Oligonucleotides For The Treatment of Muscular Dystrophy
#2677CUG REPEAT SEQUENCE BINDING AGENT
#2678METHODS AND COMPOSITIONS FOR IMPROVED TYPE I-E CRISPR BASED GENE SILENCING
#2679USE OF SBDS INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#2680Nucleic acid molecules capable of modulating target gene expression and uses thereof
#2681METHODS AND COMPOSITIONS FOR DIAGNOSIS AND TREATMENT OF CANCER
#2682Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#2683COMPOUNDS AND METHODS FOR THE TREATMENT OF CANCER
#2684METHODS AND COMPOSITIONS FOR THE TREATMENT OF CANCER OR OTHER DISEASES
#2685CAS12B SYSTEMS, METHODS, AND COMPOSITIONS FOR TARGETED DNA BASE EDITING
#2686ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA
#2687Applications of Recombined ScCas9 Enzymes for PAM-free DNA Modification
#2688RECOMBINANT POLYPEPTIDES FOR MEMBRANE FUSION AND USES THEREOF
#2689Treating metastatic cancer and model systems for metastatic disease
#2690METHODS FOR TREATING GAIN-OF-FUNCTION DISORDERS COMBINING GENE EDITING AND GENE THERAPY
#2691Treatment of primary ciliary dyskinesia with synthetic messenger RNA
#2692COMPOSITIONS AND METHODS FOR THE TREATMENT OF A BETA-CATENIN-ASSOCIATED DISEASE OR DISORDER
#2693IMPROVED DETECTION ASSAYS
#2694METHODS AND COMPOSITIONS FOR THE PRODUCTION OF XYLITOL FROM XYLOSE UTILIZING DYNAMIC METABOLIC CONTROL
#2695COMPLEXES FOR GENE DELETION AND EDITING
#2696GENETIC PHYSICAL UNCLONABLE FUNCTIONS AND METHODS OF USE THEREOF
#2697Optimized CRISPR-Cas nucleases and base editors and methods of use thereof
#2698SINGLE-STRANDED OLIGONUCLEOTIDE
#2699Modified double-stranded RNA agents
#2700ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES