109048 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
USE OF STROMAL CELL-DERIVED FACTOR 1 (SDF1) AS A BIOMARKER FOR DIAGNOSING AND TREATING SEVERE ACUTE RESPIRATORY DISTRESS SYNDROME (ARDS)
#2102COMPOSITIONS AND METHODS FOR CONTROLLING PSYLLIDS
#2103PLANT REGULATORY ELEMENTS AND USES THEREOF
#2104IHH AS A BIOMARKER AND THERAPEUTIC TARGET FOR NONALCOHOLIC STEATOHEPATITIS (NASH)
#2105COMPOSITIONS TARGETING WDR37 AND METHODS OF USE THEREOF
#2106MODULATION OF SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION 3 (STAT3) EXPRESSION
#2107MULTIPLEX EPIGENOME EDITING
#2108Incorporation of unnatural nucleotides and methods thereof
#2109RECOMBINANT EGFL7, EGFL7 ANTIBODIES, AND USES THEREOF
#2110DIAGNOSIS AND TREATMENT FOR CHRONIC INFLAMMATION AND VIRUS INFECTION
#2111EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#2112Lipids and compositions for the delivery of therapeutics
#2113ENGINEERED CELLS WITH REDUCED GENE EXPRESSION TO MITIGATE IMMUNE CELL RECOGNITION
#2114INDUCE AND ENHANCE IMMUNE RESPONSES USING RECOMBINANT REPLICON SYSTEMS
#2115RNAi APPROACH FOR CROP PEST PROTECTION
#2116ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#2117CELL PENETRATING PEPTIDE MEDIATED RNA TRANSDUCTION WITHIN INSECT CELLS
#2118VIRAL VECTOR PRODUCTION
#2119Regulatory Nucleic Acid Molecules for Enhancing Constitutive Gene Expression in Plants
#2120TRANSPOSON-BASED VECTORS AND USES
#2121Targeted trans-splicing using CRISPR/Cas13
#2122NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
#2123RNA COMPOSITIONS AND METHODS FOR INHIBITING LIPOPROTEIN(A)
#2124SIGNAL BOOST CASCADE ASSAY
#2125OLIGONUCLEOTIDES FOR PMS2 MODULATION
#2126HNF4A SARNA COMPOSITIONS AND METHODS OF USE
#2127METHODS OF GENE ASSEMBLY USING DNAZYMES AND USE IN DNA DATA STORAGE
#2128Systems, methods and compositions for sequence manipulation with optimized functional CRISPR-Cas systems
#2129METHODS AND SYSTEMS OF STRATIFYING INFLAMMATORY DISEASE PATIENTS
#2130USE OF REGULATOR OF ITPRIPL1 IN PREPARATION OF DRUG THAT REGULATES IMMUNE RESPONSES OR FIGHTS TUMORS
#2131ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES
#2132CONJUGATE GROUP AND CONJUGATE
#2133COMPOSITIONS FOR FACILITATING MEMBRANE FUSION AND USES THEREOF
#2134RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#2135MICRORNA-BASED COMPOSITIONS AND METHODS USED IN DISEASE TREATMENT
#2136COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#2137Modified ribonucleic acids and uses thereof
#2138OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
#2139Methods of Treating of Spinal Stenosis and Ligamentum Flavum Hypertrophy
#2140OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#2141MODIFIED MIR-135, CONJUGATED FORM THEREOF, AND USES OF SAME
#2142COMPOSITIONS AND METHODS FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY (FSHD)
#2143COMPOSITIONS FOR AND METHODS OF ENHANCING TISSUE REGENERATION
#2144SUPPRESSING HIPPO SIGNALING IN THE STEM CELL NICHE PROMOTES SKELETAL MUSCLE REGENERATION
#2145COMPOUNDS AND METHODS FOR MODULATING SCN2A
#2146PLASMID ADDICTION SYSTEMS
#2147NUCLEIC ACID MOLECULE FOR INDUCTION OF ASYMMETRIC RNAI FOR INHIBITING EXPRESSION OF ROR-BETA
#2148COMPOSITIONS AND METHODS FOR IMPROVED VACCINATION
#2149TREATMENTS OF NON-ALCOHOLIC STEATOHEPATITIS (NASH)
#2150LIPID NANOPARTICLE
#2151ONE-LOCUS INDUCIBLE PRECISION GUIDED STERILE INSECT TECHNIQUE OR TEMPERATURE-INDUCIBLE PRECISION GUIDED STERILE INSECT TECHNIQUE
#2152Loop-Mediated Synthetic Riboregulators
#2153CIRCULATING miRNA AND PROTEIN BIOMARKERS FOR FACIOSCAPULOHUMERAL DYSTROPHY
#2154NOVEL CRISPR ENZYMES AND SYSTEMS
#2155ADENO-ASSOCIATED VIRUS (AAV) PRODUCER CELL LINE AND RELATED METHODS
#2156EXPRESSION SYSTEM AND METHOD FOR CONTROLLING A NETWORK IN A CELL AND CELL COMPRISING THE EXPRESSION SYSTEM
#2157Compositions and methods comprising engineered short nuclear RNA (snRNA)
#2158SRNA PLATFORM FOR INHIBITING PROKARYOTIC EXPRESSION AND USE THEREOF
#2159Stabilized saRNA Compositions and Methods of Use
#2160Tuning cascade assay kinetics via molecular design
#2161MODULATING HEMATAOPOIESIS AND MYLEOID CELL PRODUCTION
#2162Agent for Regulating Expression and/or Function of RPS25 Gene
#2163COMPLEMENT FACTOR B (CFB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2164CAS9 VARIANTS AND METHODS OF USE
#2165COMPOSITION CONTAINING NUCLEIC ACID MOLECULE STABLY
#2166COMPOSITIONS AND METHODS FOR TREATING MOTOR NEURON DISEASES
#2167Genome editing method
#2168PHAGE COMPOSITIONS FOR PSEUDOMONAS COMPRISING CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF
#2169INHIBITION OF miR-29b-3p TO ENHANCE NEURONAL SURVIVAL IN HUNTINGTON'S DISEASE
#2170VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#2171SNCA IRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING SNCA-ASSOCIATED NEURODEGENERATIVE DISEASES
#2172COMPOSITIONS COMPRISING A NUCLEASE AND USES THEREOF
#2173TREATMENTS FOR RETINAL DEGENERATIVE DISEASES
#2174MODIFIED OLIGONUCLEOTIDES FOR USE IN TREATMENT OF TAUOPATHIES
#2175Compositions and Methods Using SNRNA Components
#2176METHODS AND COMPOSITIONS FOR RESTORING STMN2 LEVELS
#2177METHODS FOR ENHANCING THERAPEUTIC EFFICACY OF ISOLATED CELLS FOR CELL THERAPY
#2178METHODS AND COMPOSITIONS FOR WOUND HEALING
#2179USING DREADD FOR NEURONAL MODULATION IN TREATING NEURONAL DISEASES
#2180RNA Vectors with Hairpin-like Inserts
#2181Albumin Production and Cell Proliferation
#2182NUCLEIC ACID DUPLEXES
#2183COMPOUNDS FOR MODULATING CHMP7
#2184LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#2185SIRT1-saRNA Compositions and Methods of Use
#2186TREATMENT OF FUCHS' ENDOTHELIAL CORNEAL DYSTROPHY
#2187COMPOSITIONS AND METHODS FOR SUPPRESSING MSUTZ
#2188SYNTHETIC METHANOL INDUCIBLE PROMOTERS AND USES THEREOF
#2189COMPOSITIONS AND METHODS FOR THE DIAGNOSIS AND TREATMENT OF ITCH
#2190CASP8AP2 ANTAGONISTS FOR USE IN THE PREVENTION OR TREATMENT OF CANCER
#2191DEVELOPMENT OF NOVEL GENE THERAPEUTICS FOR INFLAMMATION-INDUCED BONE LOSS
#2192COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#2193COMPOSITIONS AND METHODS TO CONTROL INSECT PESTS
#2194ADENINE BASE EDITOR LACKING CYTOSINE EDITING ACTIVITY AND USE THEREOF
#2195GENETICALLY-MODIFIED CELLS COMPRISING A MODIFIED HUMAN T CELL RECEPTOR ALPHA CONSTANT REGION GENE
#2196APPARATUS, METHOD, AND USE FOR ULTRASOUND MEDIATED MICROBUBBLE DELIVERY OF PHARMACEUTICAL COMPOSITIONS
#2197Rotavirus vaccines
#2198Compositions and methods for nanoparticle lyophile forms
#2199Systems and methods for one-shot guide RNA (ogRNA) targeting of endogenous and source DNA
#2200ENHANCED NANOPARTICLE DELIVERY SYSTEMS
#2201bZIP TRANSCRIPTION FACTORS REGULATE CONVERSION OF NICOTINE TO NORNICOTINE
#2202MODULATION OF GENE EXPRESSION AND SCREENING FOR DEREGULATED PROTEIN EXPRESSION
#2203HUMAN ORAL MUCOSA STEM CELL SECRETOME
#2204METHODS AND COMPOSITIONS FOR INCREASED DOUBLE STRANDED RNA PRODUCTION
#2205COMPOSITIONS AND METHODS FOR INHIBITING SNCA EXPRESSION
#2206COMPOSITIONS AND METHODS FOR INHIBITING MAPT EXPRESSION
#2207METHOD OF TREATING DUCHENNE MUSCULAR DYSTROPHY
#2208COMPOSITIONS TARGETING PACS1 AND METHODS OF USE THEREOF
#2209B-SPECTRIN (SPTBN1) DEFICIENCY PROTECTS MICE FROM HIGH-FAT DIET-INDUCED LIVER DISEASE AND CANCER DEVELOPMENT
#2210VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#2211RNAi Agents for Inhibiting Expression of DUX4, Compositions Thereof, And Methods of Use
#2212MUCIN 5B (MUC5B) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2213OLIGONUCLEOTIDES FOR ATN1 MODULATION
#2214UMLILO ANTISENSE TRANSCRIPTION INHIBITORS
#2215GUIDE RNA WITH CHEMICAL MODIFICATIONS
#2216CRISPR/CAS DROPOUT SCREENING PLATFORM TO REVEAL GENETIC VULNERABILITIES ASSOCIATED WITH TAU AGGREGATION
#2217SYSTEMS FOR GENE EDITING AND METHODS OF USE THEREOF
#2218POLYPEPTIDE COMPOSITIONS COMPRISING SPACERS
#2219ANTISENSE OLIGONUCLEOTIDES AND USES THEREOF
#2220INDUCTION OF FERROPTOSIS FOR CANCER THERAPY
#2221DNA DAMAGE DEPENDENT MICRORNA SIGNATURE FOR CANCERS, METHODS AND USES RELATED THERETO
#2222Isolated Novel Nucleic Acid and Protein Molecules from Corn and Methods of Using Those Molecules to Generate Transgenic Plants with Enhanced Agronomic Traits
#2223GENETIC ELEMENTS DRIVING CIRCULAR RNA TRANSLATION AND METHODS OF USE
#2224MODIFIED RIBONUCLEIC ACIDS AND USES THEREOF
#2225Oligonucleotides conjugated to oleic acid and uses thereof
#2226USE OF MICRORNA INHIBITION TO PREVENT AND TREAT OSTEOARTHRITIS AND OTHER INFLAMMATORY DISEASES
#2227VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#2228NOVEL EFFICACIOUS MICRORNA-30C ANALOGS REDUCE APOLIPOPROTEIN B SECRETION IN HUMAN LIVER CELLS
#2229ANTISENSE OLIGOMER COMPOUNDS
#2230Methods of Rescuing Stop Codons via Genetic Reassignment with ACE-tRNA
#2231TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#2232METHODS FOR INHIBITING CHMP7 EXPRESSION IN NEURONAL CELLS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#2233BIOENGINEERED WNT5A THERAPEUTICS FOR ADVANCED CANCERS
#2234Method to Regulate ALOX12-AS1 IncRNA-Mediated Alteration of ALOX12 Protein and to Screen for Novel Drugs to Alter ALOX12 Protein Level
#2235NOVEL CRISPR-ASSOCIATED SYSTEMS AND COMPONENTS
#2236GENE THERAPY FOR ALZHEIMER'S DISEASE
#2237COMPOSITIONS AND METHODS FOR MODIFYING BACTERIAL GENE EXPRESSION
#2238PREVENTION AND/OR TREATMENT OF HEARING LOSS OR IMPAIRMENT
#2239METHODS FOR TREATING ATHEROSCLEROTIC CARDIOVASCULAR DISEASE WITH LPA-TARGETED RNAi CONSTRUCTS
#2240miR-29a-LIKE NUCLEIC ACID REAGENT, LIVER FIBROSIS INHIBITOR, AND PHARMACEUTICAL COMPOSITION
#2241Anticancer compositions and methods for making and using them
#2242Methods and compositions for genome editing in non-dividing cells
#2243COMPOSITIONS AND METHODS FOR TREATING DISEASES OF THE LIVER
#2244OPTIMIZED SIRNA SCAFFOLDS
#2245SELECTIVE RNA-MODULATING AGENTS
#2246COMPLEMENT COMPONENT C1S INHIBITORS FOR TREATING A NEUROLOGICAL DISEASE, AND RELATED COMPOSITIONS, SYSTEMS AND METHODS OF USING SAME
#2247COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#2248PEPTIDE-BASED DELIVERY OF AGENTS
#2249miRNA, and Derivative Thereof and Use Thereof
#2250METHOD FOR REGULATING GROWTH OF DECAPODA CRUSTACEANS
#2251SUMO Targeting Morpholinos as both Enhancers of Anti-Cancer Effects of Chemotherapeutic Treatments and Preventative Agents Against the Establishment of Chemoresistance
#2252Huntingtin (HTT) iRNA agent compositions and methods of use thereof
#2253NUCLEIC ACID MOLECULES WITH INCREASED GENE SILENCING ACTIVITY AND USES THEREOF
#2254COMPOSITION FOR TREATING RETINAL OR CHOROIDAL DISEASES, CONTAINING ACTA2 INHIBITOR AS ACTIVE INGREDIENT
#2255VARIANT RNAi
#2256REDUCING BETA-CATENIN EXPRESSION TO POTENTIATE IMMUNOTHERAPY
#2257MAMMALIAN CELLS FOR PRODUCING A SECRETED PROTEIN
#2258OLIGONUCLEOTIDES FOR APP MODULATION
#2259PROMOTING NUTRIENT ABSORPTION THROUGH THE COLON
#2260COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2261Methods and Compositions for Reducing Immunosupression by Tumor Cells
#2262METHODS FOR REGULATING BLOOD-CENTRAL NERVOUS SYSTEM (BLOOD-CNS) BARRIER AND USES THEREOF
#2263NOVEL RNA COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3
#2264MODIFIED FUNCTIONAL NUCLEIC ACID MOLECULES
#2265TARGETING XIST AND RNA METHYLATION FOR X REACTIVATION THERAPY
#2266PEPTIDE-BASED TRANSDUCTION OF NON-ANIONIC POLYNUCLEOTIDE ANALOGS FOR GENE EXPRESSION MODULATION
#2267PHAGE ENGINEERING: PROTECTION BY CIRCULARIZED INTERMEDIATE
#2268TYPE VI CRISPR ORTHOLOGS AND SYSTEMS
#2269NOVEL PIGGYBAC TRANSPOSON SYSTEM AND USE THEREOF
#2270PLATELETS AS DELIVERY AGENTS
#2271NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#2272METHODS AND COMPOSITIONS FOR TREATING SKELETAL MUSCULAR DYSTROPHY
#2273EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
#2274POLYMERS AND NANOPARTICLE FORMULATIONS FOR SYSTEMIC NUCLEIC ACID DELIVERY
#2275COMPOSITIONS AND METHODS FOR MODULATION OF BACTERIAL GENE EXPRESSION
#2276CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#2277Effect of Fuel Doping in ICF Targets
#2278MODULATING SYNGAP
#2279MICRORNA INHIBITOR SYSTEM AND METHODS OF USE THEREOF
#2280Compositions and Methods Targeting circ2082 for the Treatment of Cancer
#2281FOXP3S-PROMOTING MORPHOLINOS
#2282Human XIST Antisense Oligonucleotides for X Reactivation Therapy
#2283COMBINATION
#2284Mammalian cell line for protein production and library generation
#2285METHODS OF TREATING NEURONAL DISEASES USING AIMP2-DX2 AND OPTIONALLY A TARGET SEQUENCE FOR miR-142 AND COMPOSITIONS THEREOF
#2286OLIGONUCLEIC ACID CONJUGATE
#2287ENDOSOMAL ESCAPE DOMAINS FOR DELIVERY OF MACROMOLECULES INTO CELLS
#2288METHODS FOR X CHROMOSOME REACTIVATION
#2289POLYMER NANOPARTICLE, METHOD FOR THE MANUFACTURE THEREOF, AND METHOD FOR INTRACELLULAR DELIVERY OF A CARGO
#2290LIPID FORMULATIONS FOR NUCLEIC ACID DELIVERY
#2291METHODS AND COMPOSITIONS FOR MACROPHAGE POLARIZATION
#2292METHODS FOR INDUCING ADIPOSE TISSUE REMODELING USING RNAI THERAPEUTICS
#2293TARGETED GENE THERAPY FOR DM-1 MYOTONIC DYSTROPHY
#2294ABCD1 FOR TREATMENT OF NEURODISORDERS
#2295HOMOGENEOUS BETA-1,3-GLUCAN/NUCLEIC ACID COMPLEXES AND USE THEREOF
#2296SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2297USE OF SPLICE SWITCHING OLIGONUCLEOTIDES FOR EXON SKIPPING-MEDIATED KNOCKDOWN OF NF-KB COMPONENTS IN B CELLS
#2298METHODS FOR TREATING NEUROLOGICAL DISEASE
#2299TARGETED RNA EDITING BY LEVERAGING ENDOGENOUS ADAR USING ENGINEERED RNAS
#2300Tracking and Manipulating Cellular RNA via Nuclear Delivery of CRISPR/CAS9
#2301COMPOSITIONS AND METHODS OF USE OF CRISPR-CAS SYSTEMS IN NUCLEOTIDE REPEAT DISORDERS
#2302IDENTIFICATION OF PAX3-FOXO1 BINDING GENOMIC REGIONS
#2303METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#2304METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#2305Anti-transferrin receptor antibody-PMO conjugates for inducing DMD exon 44 skipping
#2306METHOD FOR DIRECT REPROGRAMMING FROM SOMATIC CELLS INTO PANCREATIC BETA CELLS BY USING MICRORNA, AND DIFFERENTIATION COMPOSITION
#2307COMPOSITIONS AND METHODS FOR MODULATING COMPLEMENT FACTOR B EXPRESSION
#2308p21 mRNA target areas for silencing
#2309COMPOUNDS AND METHODS FOR REDUCING APOE EXPRESSION
#2310BIFUNCTIONAL LENTIVIRAL VECTORS ALLOWING THE BS-GLOBIN SILENCING AND EXPRESSION OF AN ANTI-SICKLING HBB AND USES THEREOF FOR GENE THERAPY OF SICKLE CELL DISEASE
#2311PHARMACEUTICAL COMPOSITIONS COMPRISING AN ANTISENSE OLIGONUCLEOTIDE FOR ORAL ADMINISTRATION
#2312NOVEL NUCLEIC ACID MOLECULE INHIBITING EXPRESSION OF TARGET GENE
#2313PRIME EDITING GUIDE RNAS, COMPOSITIONS THEREOF, AND METHODS OF USING THE SAME
#2314USE OF LONG NON-CODING RNAS IN MEDULLOBLASTOMA
#2315Morpholinos with Increased Delivery Efficiency
#2316Nucleic acid, composition and conjugate containing same, preparation method, and use thereof
#2317RNAI AGENTS FOR HEPATITIS B VIRUS INFECTION
#2318SYSTEMS, METHODS AND COMPOSITION OF USING RNASE III MUTANTS TO PRODUCE SRNA TO CONTROL HOST PATHOGEN INFECTION
#2319METHODS AND APPARATUSES FOR BIOMOLECULE DELIVERY TO PRIMARY HUMAN HEMATOPOIETIC STEM CELLS USING NANOSTRAWS
#2320DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES
#2321RNA Interactome of Polycomb Repressive Complex 1 (PRC1)
#2322OLIGONUCLEOTIDES FOR MECP2 MODULATION
#2323DUX4 INHIBITORS AND METHODS OF USE THEREOF
#2324METHODS FOR THE REDUCTION OF Z-AAT PROTEIN LEVELS
#2325SHORT INTERFERING NUCLEIC ACID (siNA) COMPOSITIONS
#2326OLIGONUCLEOTIDES
#2327Therapeutic Bacterial Composition
#2328RNA-BASED CONTROL OF LEPIDOPTERAN PESTS
#2329Methods and compositions for transducing lymphocytes and regulating the activity thereof
#2330METHODS AND COMPOSITIONS FOR THE ACTIVATION OF GAMMA-DELTA T-CELLS
#2331Methods of Protecting RNA
#2332Modifying the specificity of plant non-coding RNA molecules for silencing gene expression
#2333Plastid-transgene-encoded nuclear gene silencing
#2334CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION
#2335MAPT RNA interference agents
#2336SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#2337METHODS FOR INTRACELLULAR DELIVERY AND ENHANCED GENE TARGETING
#2338Compounds and compositions including phosphorothioated oligodeoxynucleotide, and methods of use thereof
#2339miR-3132 upregulation of the trail pathway and apoptotic activity in cancer cells
#2340USES FOR PREVENTION OR TREATMENT OF BRAIN DISEASES USING MICRORNA
#2341REGULATION OF TRANSLATION OF EXPRESSED GENES
#2342OLIGONUCLEOTIDES FOR MLH1 MODULATION
#2343Compositions and methods of treating facioscapulohumeral muscular dystrophy
#2344SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#2345Permanent Epigenetic Gene Silencing
#2346METHODS FOR TREATING HUNTINGTON'S DISEASE
#2347Base editing of ANGPTL3 and methods of using same for treatment of disease
#2348Gene-regulating compositions and methods for improved immunotherapy
#2349LENTIVIRAL VECTOR EXPRESSING MEMBRANE-ANCHORED OR SECRETED ANTIBODY
#2350Delivery of hydrophobic active agent particles
#2351VISTA MODULATORS FOR DIAGNOSIS AND TREATMENT OF CANCER
#2352Methods for therapeutic administration of messenger ribonucleic acid drugs
#2353USE OF NOVEL MIRNA-BINDING SITE CASSETTES FOR ANTIGEN-PRESENTING CELL DETARGETING OF TRANSGENE EXPRESSION BY RAAV GENE THERAPY
#2354NUCLEIC ACIDS ENCODING CRISPR-ASSOCIATED PROTEINS AND USES THEREOF
#2355MATERIALS AND METHODS FOR THE DELIVERY OF THERAPEUTIC NUCLEIC ACIDS TO TISSUES
#2356Angelman syndrome antisense treatment
#2357TREATMENT AND DETECTION OF LIVER FIBROSIS AND LIVER DISEASE USING MICRORNA
#2358shRNA TARGETING SNORD115 LOCATIONS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN ANGELMAN SYNDROME
#2359METHODS FOR MULTIPLEXING RECOMBINASE POLYMERASE AMPLIFICATION
#2360DISCONTINUOUS OLIGONUCLEOTIDE LIGANDS
#2361IRNA COMPOSITIONS AND METHODS FOR SILENCING GROWTH FACTOR RECEPTOR BOUND PROTEIN 10 (GRB10) OR GROWTH FACTOR RECEPTOR BOUND PROTEIN 14 (GRB14) IN THE LIVER
#2362DIFFERENTIAL KNOCKOUT OF A HETEROZYGOUS ALLELE OF SAMD9
#2363BIFUNCTIONAL MOLECULES AND METHODS OF USING THEREOF
#2364ZBTB32 INHIBITORS AND USES THEREOF
#2365COMBINATION THERAPY WITH SEMAPHORIN-4D BLOCKADE AND HTT-LOWERING AGENT FOR TREATMENT OF HUNTINGTON'S DISEASE
#2366MATERIALS AND METHODS FOR TREATMENT OF FRIEDREICH ATAXIA AND OTHER RELATED DISORDERS
#2367METHODS OF TREATING AN ISCHEMIC DISEASE
#2368METHODS OF PRODUCING T REGULATORY CELLS, METHODS OF TRANSDUCING T CELLS, AND USES OF THE SAME
#2369VESICLES COMPRISING A PTEN INHIBITOR AND USES OF SAME
#2370OLIGOMERS HAVING BICYCLIC SCAFFOLD MOIETIES
#2371RNA TARGETING METHODS AND COMPOSITIONS
#2372OLIGONUCLEOTIDES TARGETING XBP1
#2373Compositions of DNA Molecules, Methods of Making Therefor, and Methods of Use Thereof
#2374METHODS AND COMPOSITIONS FOR GENOME EDITING
#2375Treatment of amyotrophic lateral sclerosis (ALS)
#2376EXOSOME SECRETED FROM GENE-MODIFIED CELLS WITH LONG NON-CODING RIBONUCLEIC ACIDS AND APPLICATION THEREOF
#2377Compositions for modulating tau expression
#2378RNAi Agents And Compositions for Inhibiting Expression of Apolipoprotein C-III (APOC3)
#2379Targeting enhancer RNAs for the treatment of primary brain tumors
#2380COMPOSITIONS AND METHOD FOR TREATING THALASSEMIA
#2381miR-17˜92 for Treatment or Protection Against Acute Kidney Injury
#2382ANTISENSE OLIGONUCLEOTIDES FOR RNA EDITING
#2383UNA OLIGOMERS FOR THE TREATMENT OF POLYGLUTAMINE DISEASES
#2384Polynucleotides containing a morpholino linker
#2385CLOSED LINEAR DNA WITH MODIFIED NUCLEOTIDES
#2386CASZ COMPOSITIONS AND METHODS OF USE
#2387Compositions and Methods of Treatment
#2388COMPOSITIONS AND METHODS FOR SIMULTANEOUSLY MODULATING EXPRESSION OF GENES
#2389METHODS AND COMPOSITIONS COMPRISING THERAPEUTIC GAMMA PEPTIDE NUCLEIC ACID-BASED MOLECULES
#2390Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
#2391MONOCLONAL ANTIBODIES TO CHEMICALLY-MODIFIED NUCLEIC ACIDS AND USES THEREOF
#2392Positional Delivery and Encoding by Oligonucleotides of Biological Cells for Single Cell Sequencing (POS SEQ)
#2393RNA COMPRISING SECRETOMES AND METHODS OF THEIR USE
#2394Compositions and Methods for Degradation of Misfolded Proteins
#2395COMPLEMENT COMPONENT 4 INHIBITORS FOR TREATING NEUROLOGICAL DISEASES, AND RELATED COMPOSITONS, SYSTEMS AND METHODS OF USING SAME
#2396MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#2397TROPHIN GENOME EDITING FOR TREATING DUCHENNE MUSCULAR DYSTROPHY (DMD)
#2398METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#2399PREPARATION METHOD FOR DIABETES EARLY WARNING AND/OR DIAGNOSTIC REAGENT KIT BASED ON HSA-MIR-320A, MEDICAMENT FOR PREVENTING DIABETES, SCREENING METHOD FOR MEDICAMENT, AND PREPARATION METHOD THEREFOR
#2400HISTIDINE-LYSINE POLYMERS AND METHODS FOR DELIVERING MRNA USING THE SAME