109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
PRODUCTS AND METHODS FOR PROMOTING MYOGENESIS
#902A NON-CANONICAL SIGNALING ACTIVITY OF CGAMP TRIGGERS DNA DAMAGE RESPONSE SIGNALING
#903ANTISENSE OLIGONUCLEOTIDES TARGETING UNC13A
#904NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#905GALNAC-MONOMERS AND GALNAC-NUCLEIC ACID CONJUGATES
#906COMPOSITIONS COMPRISING DOPED SILICON PARTICLES, AND RELATED METHODS
#907NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF
#908MODULATORS OF ENaC EXPRESSION
#909MODIFIED OLIGONUCLEOTIDES TARGETING SNPs
#910METHODS FOR REACTIVATING GENES ON THE INACTIVE X CHROMOSOME
#911LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE
#912NUCLEIC ACID CONSTRUCT ENABLING EXPRESSION AND INHIBITION OF GENE SIMULTANEOUSLY
#913CONJUGATE OF SAPONIN, OLIGONUCLEOTIDE AND GALNAC
#914BLOCK COPOLYMERS
#915Therapeutic Compounds for Inhibiting and Reducing the Expression of Cell Surface Proteins
#916TOPICAL DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#917CELLULAR THERAPIES FOR CANCER BY INHIBITION OF MONOCARBOXYLATE TRANSPORTER 11
#918COMPOSITIONS AND METHODS FOR TREATMENT OF GAUCHER DISEASE
#919NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING SAME, AND PREPARATION METHOD AND USE
#920TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#921LIPID NANOPARTICLE COMPOSITIONS FOR DELIVERY OF MRNA AND LONG NUCLEIC ACIDS
#922METHOD FOR RNAI FUNGICIDE GENERATING AND THE RNAI FUNGICIDE THEREOF
#923PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#924Multi-Valent Oligonucleotide Agent and Methods of Use Thereof
#925METHOD FOR PRODUCING DIRECTLY REPROGRAMMED NATURAL KILLER CELLS AND USES THEREOF
#926NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#927COMPOSITIONS AND METHODS FOR ENHANCING THE THERAPEUTIC POTENTIAL OF STEM CELLS
#928MITOCHONDRIAL SUPERCOMPLEX FORMATION PROMOTER, COMPOSITION FOR MAINTAINING OR IMPROVING MUSCULAR STRENGTH, THERAPEUTIC OR PREVENTATIVE PHARMACEUTICAL COMPOSITION FOR DISEASES WHICH DECREASE MITOCHONDRIAL FUNCTION OR MUSCULAR FUNCTION, AND SCREENING METHOD FOR SUBSTANCES WHICH CONTRIBUTE TO FORMATION OF MITOCHONDRIAL SUPERCOMPLEX
#929ANTI-FIBROSIS PHARMACEUTICAL COMPOSITION AND APPLICATION THEREOF
#930TRACKING APOBEC MUTATIONAL SIGNATURES IN TUMOR CELLS
#931COMPOSITIONS AND METHODS FOR INHIBITING TRANSMEMBRANE SERINE PROTEASE 6 (TMPRSS6) EXPRESSION
#932TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#933COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#934INVERTED CHIMERIC siRNA MOLECULES AND METHODS OF USE THEREOF
#935SMALL INTERFERING RNA TARGETING HBV AND USES THEREOF
#936COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#937CTLA-4 APTAMER CONJUGATES
#938DOUBLE-STRANDED OLIGONUCLEOTIDE, COMPOSITION AND CONJUGATE CONTAINING DOUBLE-STRANDED OLIGONUCLEOTIDE, AND PREPARATION METHODS AND USES
#939STABILIZATION OF OLIGONUCLEOTIDE AND OLIGONUCLEOTIDE-PROTEIN COMPLEX USING ALKYLATED PHOSPHATE
#940METHODS AND COMPOSITIONS TO DIAGNOSE AND TREAT TAUOPATHIES UTILIZING TRANSCRIPT VARIANTS OF PSEN2
#941METABOLIC DISORDER-ASSOCIATED TARGET GENE IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#942METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS
#943USE OF A LRP1 INHIBITOR IN TREATING NOTCH SIGNALING-DEPENDENT DISEASE
#944Inhibition of Diacylglycerol Kinase to Augment Adoptive T cell Transfer
#945METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY TARGETING AXL SIGNALING
#946CHEMICALLY MODIFIED OLIGONUCLEOTIDES
#947LEUCINE-RICH REPEAT KINASE 2 (LRRK2) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#948METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER
#949UNA AMIDITES AND USES THEREOF
#950OLIGONUCLEOTIDES FOR HTT-1A MODULATION
#951COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)
#952OLIGONUCLEOTIDE CONJUGATES TARGETED TO THE TRANSFERRIN RECEPTOR
#953NATURAL KILLER CELLS ENGINEERED TO REDUCE OR ELIMINATE CBL-B AND USES THEREOF
#954AGENT FOR USE IN THE TREATMENT OF GLIOMA
#955NOVEL REDOX-BASED THERAPEUTIC APPROACH FOR TREATMENT OF CANCER
#956METHODS AND COMPOSITIONS TO TREAT HUNTINGTON'S DISEASE BY TARGETING ALOX5- MEDIATED FERROPTOSIS
#957LIPID NANOPARTICLES AND METHOD FOR PREPARING SAME
#958METHOD FOR IMPROVING GENETIC ENGINEERING OF ADOPTIVE CELL THERAPIES
#959Method of Treatment for Auditory Dysfunction
#960MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING POMPE DISEASE
#961MODULATION OF NOX4 EXPRESSION
#962FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE WOUND HEALING
#963COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#964INSULIN-LIKE GROWTH FACTOR BINDING PROTEIN, ACID LABILE SUBUNIT (IGFALS) AND INSULIN-LIKE GROWTH FACTOR 1 (IGF-1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#965SELECTIVE DELIVERY OF OLIGONUCLEOTIDES TO GLIAL CELLS
#966ENGINEERED NATURAL KILLER (NK) CELLS AND COMPOSITIONS AND METHODS THEREOF
#967CHLORELLA-BASED PRODUCTION OF EXTRACELLULAR VESICLE-EMBEDDED SMALL RNAS FOR BIOCONTROL APPLICATIONS
#968COMPOSITIONS AND METHODS FOR MODULATING CANCER IMMUNE FITNESS
#969COMPOSITIONS FOR TREATING AND/OR PREVENTING CELL OR TISSUE NECROSIS SPECIFICALLY TARGETING CATHEPSIN C AND/OR CELA1 AND/OR CELA3A AND/OR STRUCTURALLY RELATED ENZYMES THERETO
#970Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of use thereof to target dystrophin and to treat Duchenne muscular dystrophy
#971CARBOHYDRATE CONJUGATES FOR THE DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#972BRANCHED OLIGONUCLEOTIDES
#973METHODS FOR DIAGNOSIS AND TREATMENT OF TYPE 1 DIABETES
#974CONTROL OF PLANT PESTS USING RNA MOLECULES
#975COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM
#976COMPOSITIONS AND METHODS FOR TREATING CANCER
#977GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#978TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#979COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#980TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS
#981TREATMENT OF MTRES1 RELATED DISEASES AND DISORDERS
#982TREATMENT OF PLIN1 RELATED DISEASES AND DISORDERS
#983RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#984OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION
#985THERAPEUTIC AGENT FOR MUSCULAR ATROPHY
#986COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#987COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#988Compositions And Methods For Enhancing Immunotherapy
#989COMPOSITIONS AND METHODS OF TREATING DISEASES ASSOCIATED WITH BILE ACID TRANSPORTER
#990TREATMENT OF ANGPTL4 RELATED DISEASES
#991HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#992Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors
#993DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#994LIGAND-BINDING NUCLEIC ACID COMPLEX
#995FOLLICULIN iRNA COMPOSITIONS AND METHODS THEREOF
#996RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#997METHOD FOR IMMORTALISING VESICLE-SECRETING CELLS
#998METHODS AND COMPOSITIONS FOR MODIFYING MACROPHAGE POLARIZATION INTO PRO-INFLAMMATORY CELLS TO TREAT CANCER
#999CD71 BINDING FIBRONECTIN TYPE III DOMAINS
#1000SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1001POLYNUCLEIC ACID MOLECULES TARGETING PCSK9 AND USES THEREOF
#1002COMPOSITIONS AND METHODS FOR THE INHIBITION OF NERVE GROWTH FACTOR AND THE TREATMENT/PREVENTION OF ATRIAL FIBRILLATION
#1003COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF HEPATITIS B VIRUS (HBV)PROTEIN
#1004METHODS AND COMPOSITIONS FOR MODULATING STING SIGNALING AND INNATE IMMUNE RESPONSES
#1005Asymmetric Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#1006COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1007KRAB-Containing Zinc Finger Protein And Cancer
#1008METHODS AND COMPOSITIONS FOR CELL REPROGRAMMING
#1009COMPOSITIONS AND METHODS FOR TRANSGENE EXPRESSION
#1010NANOPARTICLE COMPRISING PEPTIDE-LIPID CONJUGATE FOR DELIVERING OLIGONUCLEOTIDE INTO TARGET CELL AND PHARMACEUTICAL COMPOSITION COMPRISING SAME
#1011COMBINATION OF A TLR8 MODULATING COMPOUND AND ANTI-HBV siRNA THERAPEUTICS
#1012COMPOSITION FOR TREATING METASTATIC SOLID CANCER, COMPRISING TSG6 INHIBITOR
#1013MODULAR LIPID COMPOUNDS AND TWO- TO THREE-COMPONENT LIPID NANOPARTICLE COMPOSITIONS
#1014SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
#1015Methods and Compositions for Determining pH
#1016COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#1017BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1018Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#1019COMPOSITIONS AND METHODS OF TARGETING THE PAX6 SIGNALING PATHWAY TO REDUCE FORMATION OF AMYLOID BETA PLAQUES AND NEUROFIBRILLARY TANGLES
#1020MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1021COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#1022SIRNAS TARGETING SLC10A1 TRANSCRIPTS, COMPOSITIONS AND USES THEREOF
#1023METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#1024RABIES VIRAL GLYCOPROTEIN COMPOSITIONS AND METHODS OF USE
#1025PRE-IMMUNIZATION AND IMMUNOTHERAPY
#1026COMPOSITIONS AND METHODS FOR PROMOTING THE MINERALIZATION OF BIOLOGICAL TISSUE
#1027FATTY ACID CONJUGATES OF NUCLEIC ACIDS
#1028RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#1029Treatment Of Stroke With 1,4-Alpha-Glucan-Branching Enzyme (GBE1) Inhibitors
#1030METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#1031POLYNUCLEOTIDE CONSTRUCTS
#1032CATIONIC LIPIDS FOR NUCLEIC ACID DELIVERY AND PREPARATION THEREOF
#1033TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#1034METHODS OF USING USP15 INHIBITORS
#1035COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#1036INHIBITORS OF MITOFERRIN-2 FOR USE IN TREATING CANCER
#1037HOST FACTORS THAT ENHANCE VIRAL PRODUCTION VIA VIRALLY DRIVEN FITNESS-BASED CRISPR SCREENING
#1038HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1039SIRNA CONSTRUCTS FOR INHIBITING GENE EXPRESSION IN TARGETED CANCER CELLS
#1040MULTITARGETING RNA COMPOSITIONS
#1041PREVENTION OR TREATMENT OF MYOPATHY USING MIR-33B INHIBITOR
#1042Muscle targeting complexes and uses thereof for treating myotonic dystrophy
#1043HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#1044IN-SITU CRYO-IMMUNE ENGINEERING FOR CANCER IMMUNOTHERAPY
#1045METHODS OF TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS
#1046Methods and Compositions for Treating, Ameliorating, and/or Preventing Chronic Kidney Disease (CKD) and Complications thereof by Regulating DPEP1, CASP9, ACSS2 and/or FASN
#1047ALLELE-SPECIFIC SILENCING THERAPY FOR DYNAMIN 2-RELATED DISEASES
#1048LIPID NANOPARTICLES AND METHODS OF USE
#1049Compositions for Inhibiting Growth of Targeted Cells
#1050Multitargeting RNA Immunotherapy Compositions
#1051COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#1052NUCLEIC ACID DELIVERY SYSTEM AND APPLICATION THEREOF
#1053CHIRAL CONTROL
#1054siRNA AND USE THEREOF
#1055VON WILLEBRAND FACTOR (VWF) INHIBITORS
#1056TM4SF19 INHIBITOR AND USES THEREOF
#1057METHODS AND COMPOSITIONS FOR REDUCING NUCLEIC ACID VECTOR-INDUCED TOXICITY IN THE INNER EAR
#1058COMPOSITION FOR TREATING OSTEOARTHRITIS
#1059METHOD OF TREATING BREAST CANCER IN A SUBJECT BY INHIBITING TUBB2B
#1060COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS
#1061COLON CANCER-SPECIFIC TARGET EXOSOME COMPOSITION AS DRUG DELIVERY MATERIAL, AND USE THEREOF
#1062REPROGRAMMING OF NON-NEURONAL CELLS INTO NEURONS AND METHODS AND COMPOSITIONS TO TREAT NEURODEGENERATIVE DISEASES AND DISORDERS
#1063CHITOSAN-CONTAINING NANOPARTICLES FOR DELIVERY OF POLYNUCLEOTIDES
#1064COMPOSITIONS AND METHODS FOR TARGETED DELIVERY TO CELLS
#1065COMPOSITIONS FOR TREATING HEART DISEASE BY INHIBITING THE ACTION OF mAKAP-beta
#1066METHOD OF TREATING BREAST CANCER IN A SUBJECT BY INHIBITING TUBB2B
#1067INHIBITOR OF SUV39H1 HISTONE METHYLTRANSFERASE FOR USE IN CANCER COMBINATION THERAPY
#1068METHODS AND USES OF PROTEIN DISULFIDE ISOMERASE INHIBITORY COMPOUNDS
#1069iRNA COMPOSITIONS AND METHODS FOR SILENCING CHITINASE 3-LIKE PROTEIN 1/YKL-40 (CHI3L1/YKL-40) PROTEIN
#1070ELONGATION OF VERY LONG CHAIN FATTY ACIDS PROTEIN 1 (ELOVL1) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1071METHODS OF MODULATING ALK
#1072INHIBITORY NUCLEIC ACIDS FOR FACTOR H FAMILY PROTEINS
#1073DNA CONSTRUCTS COMPRISING ALTERNATIVE PROMOTERS
#1074TARGETING PIEZO1 TO TREAT INHERITED AND AGE-RELATED MACULAR DEGENERATIONS
#1075ORAL DELIVERY OF OLIGONUCLEOTIDES
#1076SUBSTRATE SEQUENCE DESIGN WORKFLOW FOR THE RNAI-MEDIATED MULTI-SITE REGULATION OF GENOMIC AND SUB-GENOMIC VIRAL RNAS
#1077METHODS OF DETECTING AND REDUCING CANCER CELL CENTRAL NERVOUS SYSTEM COLONIZATION
#1078USE OF ODORANT RECEPTOR FOR SUPPRESSING LACTATE-INDUCED M2-TYPE DIFFERENTIATION OF TUMOR-ASSOCIATED MACROPHAGES AND TUMOR GROWTH
#1079NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE
#1080DIAGNOSTIC DEVICE FOR LOCAL INTRAVENOUS BIOMARKER MEASUREMENTS AND METHODS OF USE THEREOF
#1081Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors
#1082STEAROYL-COA DESATURASE 5 (SCD5) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1083NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#1084ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1085METHOD AND COMPOSITIONS FOR PREVENTING TUMOR DEVELOPMENT AND METASTASIS
#1086MICROGLIAL GENE SILENCING USING DOUBLE-STRANDED SIRNA
#1087TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#1088NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#1089TISSUE-SPECIFIC NUCLEIC ACID DELIVERY BY MIXED CATIONIC LIPID PARTICLES
#1090DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES
#1091BIOMARKERS OF AGING FOR DETECTION AND TREATMENT OF DISORDERS
#1092ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1093COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION
#1094CONJUGATES OF SIRNA AND ANTISENSE OLIGONUCLEOTIDES (SIRNASO) AND METHODS OF USE IN GENE SILENCING
#1095Use of CD56 to predict the differentiation potential of muscle stem cells
#1096METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES
#1097NOVEL PEPTIDE-OLIGONUCLEOTIDE CONJUGATE AND USE THEREOF
#1098MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#1099H-1 PV EXPRESSING RNAi EFFECTORS
#1100TRANSMEMBRANE PROTEASE, SERINE 6 (TMPRSS6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1101OLIGONUCLEOTIDES TARGETING S6K1
#1102KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1103VARIANT RNAi
#1104Non-liposomal systems for nucleic acid delivery
#1105INHIBITION OF FGR REDUCES FIBROSIS
#1106DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS
#1107CALCIUM VOLTAGE-GATED CHANNEL AUXILIARY SUBUNIT GAMMA 1 (CACNG1) BINDING PROTEINS AND CACNG1-MEDIATED DELIVERY TO SKELETAL MUSCLE
#1108STAUFEN1 AGENTS AND ASSOCIATED METHODS
#1109COMPOSITIONS AND METHODS FOR TREATING HYPERCHOLESTEROLEMIA
#1110FN3 DOMAIN-SIRNA CONJUGATES AND USES THEREOF
#1111COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PCSK9
#1112TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#1113ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1114DOSING OF siRNA COMPOUNDS TO THE CISTERNA MAGNA
#1115ANTI-C5 ANTIBODY/C5 IRNA CO-FORMULATIONS AND COMBINATION THERAPIES
#1116DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES
#1117GalNAc compositions for improving siRNA bioavailability
#1118RUNX1 Inhibition for Treatment of Proliferative Vitreoretinopathy and Conditions Associated with Epithelial to Mesenchymal Transition
#1119Skeletal Muscle Delivery Platforms and Methods of Use
#1120OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1121COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1122Cationic sulfonamide amino lipids and amphiphilic zwitterionic amino lipids
#1123COMPOSITIONS AND METHODS FOR FIBROBLAST GROWTH FACTOR RECEPTOR 3-MEDIATED DELIVERY TO ASTROCYTES
#1124LOSS OF LIPID KINASE PI5P4K GAMMA RESTRICTS TUMOR GROWTH
#1125CANCER THERAPY
#1126RNAi agents for inhibiting expression of complement component C3 (C3), pharmaceutical compositions thereof, and methods of use
#1127METHODS AND COMPOSITIONS FOR ACCELERATING OLIGODENDROCYTE MATURATION
#1128TEMPLATE DIRECTED IMMUNOMODULATION FOR CANCER THERAPY
#1129METHOD FOR PRODUCING HEMATOPOIETIC CELLS FROM STEM CELLS USING VASCULAR ORGANOIDS
#1130COMPOSITIONS AND METHODS FOR INHIBITION OF CELL-PENETRATING ANTIBODIES
#1131NON-VIRAL GENE/CARRIER COMPLEX FOR PREVENTION OR TREATMENT OF ACUTE INFLAMMATORY DISEASE
#1132KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1133NUCLEOSIDE CONTAINING siRNAS FOR TREATING VIRAL DISEASES
#1134METHOD OF TREATING FATTY LIVER DISEASE
#1135NUCLEIC ACIDS SIMULTANEOUSLY INHIBITING EXPRESSION OF C-MET GENE AND PD-L1 GENE
#1136METHODS AND COMPOSITIONS USED TO MODIFY CHROMATIN ARCHITECTURE TO REGULATE PHENOTYPE IN AGING AND CANCER
#1137METHODS OF RESTORING FUNCTIONAL CAPACITY AND LINEAGE COMPOSITION OF AN AGING BLOOD AND VASCULAR SYSTEM
#1138METHODS OF DELIVERING ANIONIC AGENTS IN VIVO USING NON-VIRAL NANOPARTICLE-BASED DELIVERY SYSTEMS
#1139A SIRNA DRUG, A PHARMACEUTICAL COMPOSITION, A SIRNA-SMALL MOLECULE DRUG CONJUGATE, AND THE APPLICATION THEREOF
#1140KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1141METHODS FOR THE TREATMENT OF NASH WITH ADVANCED FIBROSIS AND/OR CIRRHOSIS
#1142SUPEROXIDE DISMUTASE 1 (SOD1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING SUPEROXIDE DISMUTASE 1- (SOD1-) ASSOCIATED NEURODEGENERATIVE DISEASES
#1143MULTI-CONJUGATE OF SIRNA AND PREPARING METHOD THEREOF
#1144MODULATING REGULATORY T CELL FUNCTION IN AUTOIMMUNE DISEASE AND CANCER
#1145Lipid formulations for delivery of therapeutic agents
#1146TREATING DISORDERS ASSOCIATED WITH DYRK1A DYSFUNCTION
#1147PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1148Compositions and methods for organ specific delivery of nucleic acids
#1149VIRAL VECTOR-BASED RNA DELIVERY SYSTEM AND USE THEREOF
#1150GENE CIRCUIT, RNA DELIVERY SYSTEM AND USE THEREOF
#1151SOLUTE CARRIER FAMILY MEMBER IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1152METHODS AND COMPOSITIONS FOR MODULATING PLASMINOGEN
#1153SIRNAS AGAINST KRAS AND RAF1
#1154CHAPERONIN-CONTAINING TCP-1 INHIBITORS FOR THE TREATMENT OF CANCER
#1155ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE
#1156ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT
#1157RNA DELIVERY SYSTEM FOR TREATMENT OF HUNTINGTON'S DISEASE
#1158CD70-TARGETED MICELLES ENHANCE HIF2? siRNA DELIVERY AND INHIBIT ONCOGENIC FUNCTIONS IN PATIENT-DERIVED CLEAR CELL RENAL CARCINOMA CELLS
#1159RNA PLASMID DELIVERY SYSTEM AND APPLICATION THEREOF
#1160RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE
#1161HSD17B13 VARIANTS AND USES THEREOF
#1162MODIFICATION OF IMMUNE CELLS FOR REDUCING TOXICITY AND USES THEREOF IN ADOPTIVE CELL THERAPY
#1163METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS
#1164TREATMENT AND DIAGNOSIS OF IMMUNE DISORDERS
#1165Factor XII (F12) iRNA compositions and methods of use thereof
#1166GLYCOGEN SYNTHASE KINASE 3 ALPHA (GSK3 ALPHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1167OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1168COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#1169MODIFIED OLIGONUCLEOTIDES TARGETING SNPs
#1170MODULATION OF TRANSTHYRETIN EXPRESSION
#1171TM4SF19 INHIBITOR AND USES THEREOF
#1172METHOD OF TREATMENT OF MALARIA BY TARGETTING OPEN READING FRAMES
#1173METHODS AND COMPOSITIONS FOR REDUCING NUCLEIC ACID VECTOR-INDUCED TOXICITY IN THE INNER EAR
#1174PEPTIDIC BLOCKS FOR NUCLEIC ACID DELIVERY
#1175CATIONIC AMPHIPHILIC POLYMERS FOR CODELIVERY OF HYDROPHOBIC AGENTS AND NUCLEIC ACIDS
#1176PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1177Diagnostic kit for metastasis and invasion of breast cancer and use of shRNA molecule for silencing expression of human LINC01614
#1178RNAI AGENT FOR INHIBITING HBV EXPRESSION AND USE THEREOF
#1179RNA CLEAVAGE-INDUCED TRANSCRIPT STABILIZER AND USES THEREOF
#1180COMPOUNDS FOR TREATMENT OF OSTEOARTHRITIS
#1181Lipid-pegylated compounds, preparations and uses thereof
#1182COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF GENES
#1183METHODS AND COMPOSITIONS FOR DIAGNOSING AND TREATING PROSTATE CANCER BASED ON LONG NONCODING RNA OVERLAPPING THE LCK GENE THAT REGULATES PROSTATE CANCER CELL GROWTH
#1184LIPOPROTEIN-MIMICKING SOLID LIPID NANOPARTICLES FOR DRUG DELIVERY AND USES THEREOF
#1185COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF GENES
#1186iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)
#1187MODIFIED OLIGONUCLEOTIDES
#1188COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#1189A JMJD6 TARGETING AGENT FOR TREATING PROSTATE CANCER
#1190Advanced Cell-Permeable Peptide Carriers
#1191PREVENTION AND/OR TREATMENT OF INFLAMMATORY SKIN DISEASE
#1192METHODS FOR PROPHYLACTIC AND THERAPEUTIC TREATMENT OF 2019-nCoV USING siRNAs AGAINST ORF1AB and N-Protein
#1193COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES
#1194OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1195COMBINATION siRNA AND PEPTIDE DOCKING VEHICLE (PDoV) COMPOSITIONS AND METHODS OF THEIR USE FOR IMPROVED REGULATION AND FUNCTIONALITY
#1196METHODS FOR TREATING AND AMELIORATING CANCER
#1197PRE-IMMUNIZATION AND IMMUNOTHERAPY
#1198METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY
#1199COMPOSITION COMPRISING EMP3 INHIBITOR FOR INHIBITING GROWTH OF CANCER STEMCELL AND USE THEREOF
#1200OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF