ClassID:

109145

C12N2310/14 - page 4 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.

Recent Application in this class:
#901
20240335505
2024-10-10

PRODUCTS AND METHODS FOR PROMOTING MYOGENESIS

#902
20240335465
2024-10-10

A NON-CANONICAL SIGNALING ACTIVITY OF CGAMP TRIGGERS DNA DAMAGE RESPONSE SIGNALING

#903
20240327845
2024-10-03

ANTISENSE OLIGONUCLEOTIDES TARGETING UNC13A

#904
20240327843
2024-10-03

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL

#905
20240327842
2024-10-03

GALNAC-MONOMERS AND GALNAC-NUCLEIC ACID CONJUGATES

#906
20240327841
2024-10-03

COMPOSITIONS COMPRISING DOPED SILICON PARTICLES, AND RELATED METHODS

#907
20240327839
2024-10-03

NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF

#908
20240327838
2024-10-03

MODULATORS OF ENaC EXPRESSION

#909
20240327836
2024-10-03

MODIFIED OLIGONUCLEOTIDES TARGETING SNPs

#910
20240327835
2024-10-03

METHODS FOR REACTIVATING GENES ON THE INACTIVE X CHROMOSOME

#911
20240327834
2024-10-03

LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE

#912
20240327832
2024-10-03

NUCLEIC ACID CONSTRUCT ENABLING EXPRESSION AND INHIBITION OF GENE SIMULTANEOUSLY

#913
20240327829
2024-10-03

CONJUGATE OF SAPONIN, OLIGONUCLEOTIDE AND GALNAC

#914
20240325552
2024-10-03

BLOCK COPOLYMERS

#915
20240325550
2024-10-03

Therapeutic Compounds for Inhibiting and Reducing the Expression of Cell Surface Proteins

#916
20240325546
2024-10-03

TOPICAL DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES

#917
20240325537
2024-10-03

CELLULAR THERAPIES FOR CANCER BY INHIBITION OF MONOCARBOXYLATE TRANSPORTER 11

#918
20240325506
2024-10-03

COMPOSITIONS AND METHODS FOR TREATMENT OF GAUCHER DISEASE

#919
20240325428
2024-10-03

NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING SAME, AND PREPARATION METHOD AND USE

#920
20240325427
2024-10-03

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#921
20240325315
2024-10-03

LIPID NANOPARTICLE COMPOSITIONS FOR DELIVERY OF MRNA AND LONG NUCLEIC ACIDS

#922
20240324602
2024-10-03

METHOD FOR RNAI FUNGICIDE GENERATING AND THE RNAI FUNGICIDE THEREOF

#923
20240318184
2024-09-26

PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#924
20240318174
2024-09-26

Multi-Valent Oligonucleotide Agent and Methods of Use Thereof

#925
20240318139
2024-09-26

METHOD FOR PRODUCING DIRECTLY REPROGRAMMED NATURAL KILLER CELLS AND USES THEREOF

#926
20240316206
2024-09-26

NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS

#927
20240316111
2024-09-26

COMPOSITIONS AND METHODS FOR ENHANCING THE THERAPEUTIC POTENTIAL OF STEM CELLS

#928
20240316052
2024-09-26

MITOCHONDRIAL SUPERCOMPLEX FORMATION PROMOTER, COMPOSITION FOR MAINTAINING OR IMPROVING MUSCULAR STRENGTH, THERAPEUTIC OR PREVENTATIVE PHARMACEUTICAL COMPOSITION FOR DISEASES WHICH DECREASE MITOCHONDRIAL FUNCTION OR MUSCULAR FUNCTION, AND SCREENING METHOD FOR SUBSTANCES WHICH CONTRIBUTE TO FORMATION OF MITOCHONDRIAL SUPERCOMPLEX

#929
20240316011
2024-09-26

ANTI-FIBROSIS PHARMACEUTICAL COMPOSITION AND APPLICATION THEREOF

#930
20240309457
2024-09-19

TRACKING APOBEC MUTATIONAL SIGNATURES IN TUMOR CELLS

#931
20240309388
2024-09-19

COMPOSITIONS AND METHODS FOR INHIBITING TRANSMEMBRANE SERINE PROTEASE 6 (TMPRSS6) EXPRESSION

#932
20240309387
2024-09-19

TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#933
20240309386
2024-09-19

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE

#934
20240309384
2024-09-19

INVERTED CHIMERIC siRNA MOLECULES AND METHODS OF USE THEREOF

#935
20240309383
2024-09-19

SMALL INTERFERING RNA TARGETING HBV AND USES THEREOF

#936
20240309382
2024-09-19

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#937
20240309379
2024-09-19

CTLA-4 APTAMER CONJUGATES

#938
20240309378
2024-09-19

DOUBLE-STRANDED OLIGONUCLEOTIDE, COMPOSITION AND CONJUGATE CONTAINING DOUBLE-STRANDED OLIGONUCLEOTIDE, AND PREPARATION METHODS AND USES

#939
20240309372
2024-09-19

STABILIZATION OF OLIGONUCLEOTIDE AND OLIGONUCLEOTIDE-PROTEIN COMPLEX USING ALKYLATED PHOSPHATE

#940
20240309371
2024-09-19

METHODS AND COMPOSITIONS TO DIAGNOSE AND TREAT TAUOPATHIES UTILIZING TRANSCRIPT VARIANTS OF PSEN2

#941
20240309370
2024-09-19

METABOLIC DISORDER-ASSOCIATED TARGET GENE IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#942
20240307534
2024-09-19

METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS

#943
20240307489
2024-09-19

USE OF A LRP1 INHIBITOR IN TREATING NOTCH SIGNALING-DEPENDENT DISEASE

#944
20240307445
2024-09-19

Inhibition of Diacylglycerol Kinase to Augment Adoptive T cell Transfer

#945
20240307390
2024-09-19

METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY TARGETING AXL SIGNALING

#946
20240301430
2024-09-12

CHEMICALLY MODIFIED OLIGONUCLEOTIDES

#947
20240301426
2024-09-12

LEUCINE-RICH REPEAT KINASE 2 (LRRK2) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#948
20240301425
2024-09-12

METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER

#949
20240301419
2024-09-12

UNA AMIDITES AND USES THEREOF

#950
20240301410
2024-09-12

OLIGONUCLEOTIDES FOR HTT-1A MODULATION

#951
20240301406
2024-09-12

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)

#952
20240299575
2024-09-12

OLIGONUCLEOTIDE CONJUGATES TARGETED TO THE TRANSFERRIN RECEPTOR

#953
20240299542
2024-09-12

NATURAL KILLER CELLS ENGINEERED TO REDUCE OR ELIMINATE CBL-B AND USES THEREOF

#954
20240299538
2024-09-12

AGENT FOR USE IN THE TREATMENT OF GLIOMA

#955
20240299401
2024-09-12

NOVEL REDOX-BASED THERAPEUTIC APPROACH FOR TREATMENT OF CANCER

#956
20240299347
2024-09-12

METHODS AND COMPOSITIONS TO TREAT HUNTINGTON'S DISEASE BY TARGETING ALOX5- MEDIATED FERROPTOSIS

#957
20240299301
2024-09-12

LIPID NANOPARTICLES AND METHOD FOR PREPARING SAME

#958
20240294943
2024-09-05

METHOD FOR IMPROVING GENETIC ENGINEERING OF ADOPTIVE CELL THERAPIES

#959
20240294925
2024-09-05

Method of Treatment for Auditory Dysfunction

#960
20240294921
2024-09-05

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING POMPE DISEASE

#961
20240294920
2024-09-05

MODULATION OF NOX4 EXPRESSION

#962
20240294918
2024-09-05

FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE WOUND HEALING

#963
20240294912
2024-09-05

COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#964
20240294911
2024-09-05

INSULIN-LIKE GROWTH FACTOR BINDING PROTEIN, ACID LABILE SUBUNIT (IGFALS) AND INSULIN-LIKE GROWTH FACTOR 1 (IGF-1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#965
20240294907
2024-09-05

SELECTIVE DELIVERY OF OLIGONUCLEOTIDES TO GLIAL CELLS

#966
20240294874
2024-09-05

ENGINEERED NATURAL KILLER (NK) CELLS AND COMPOSITIONS AND METHODS THEREOF

#967
20240294864
2024-09-05

CHLORELLA-BASED PRODUCTION OF EXTRACELLULAR VESICLE-EMBEDDED SMALL RNAS FOR BIOCONTROL APPLICATIONS

#968
20240294643
2024-09-05

COMPOSITIONS AND METHODS FOR MODULATING CANCER IMMUNE FITNESS

#969
20240294480
2024-09-05

COMPOSITIONS FOR TREATING AND/OR PREVENTING CELL OR TISSUE NECROSIS SPECIFICALLY TARGETING CATHEPSIN C AND/OR CELA1 AND/OR CELA3A AND/OR STRUCTURALLY RELATED ENZYMES THERETO

#970
20240293568
2024-09-05

Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of use thereof to target dystrophin and to treat Duchenne muscular dystrophy

#971
20240293555
2024-09-05

CARBOHYDRATE CONJUGATES FOR THE DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES

#972
20240293550
2024-09-05

BRANCHED OLIGONUCLEOTIDES

#973
20240293473
2024-09-05

METHODS FOR DIAGNOSIS AND TREATMENT OF TYPE 1 DIABETES

#974
20240292845
2024-09-05

CONTROL OF PLANT PESTS USING RNA MOLECULES

#975
20240287526
2024-08-29

COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM

#976
20240287525
2024-08-29

COMPOSITIONS AND METHODS FOR TREATING CANCER

#977
20240287524
2024-08-29

GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#978
20240287523
2024-08-29

TREATMENT OF MST1 RELATED DISEASES AND DISORDERS

#979
20240287522
2024-08-29

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#980
20240287519
2024-08-29

TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS

#981
20240287518
2024-08-29

TREATMENT OF MTRES1 RELATED DISEASES AND DISORDERS

#982
20240287517
2024-08-29

TREATMENT OF PLIN1 RELATED DISEASES AND DISORDERS

#983
20240287515
2024-08-29

RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)

#984
20240287514
2024-08-29

OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION

#985
20240287173
2024-08-29

THERAPEUTIC AGENT FOR MUSCULAR ATROPHY

#986
20240285775
2024-08-29

COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS

#987
20240285774
2024-08-29

COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS

#988
20240285683
2024-08-29

Compositions And Methods For Enhancing Immunotherapy

#989
20240279667
2024-08-22

COMPOSITIONS AND METHODS OF TREATING DISEASES ASSOCIATED WITH BILE ACID TRANSPORTER

#990
20240279663
2024-08-22

TREATMENT OF ANGPTL4 RELATED DISEASES

#991
20240279661
2024-08-22

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

#992
20240279660
2024-08-22

Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors

#993
20240279658
2024-08-22

DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO

#994
20240279655
2024-08-22

LIGAND-BINDING NUCLEIC ACID COMPLEX

#995
20240279653
2024-08-22

FOLLICULIN iRNA COMPOSITIONS AND METHODS THEREOF

#996
20240279652
2024-08-22

RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES

#997
20240279610
2024-08-22

METHOD FOR IMMORTALISING VESICLE-SECRETING CELLS

#998
20240279352
2024-08-22

METHODS AND COMPOSITIONS FOR MODIFYING MACROPHAGE POLARIZATION INTO PRO-INFLAMMATORY CELLS TO TREAT CANCER

#999
20240277858
2024-08-22

CD71 BINDING FIBRONECTIN TYPE III DOMAINS

#1000
20240271144
2024-08-15

SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1001
20240271143
2024-08-15

POLYNUCLEIC ACID MOLECULES TARGETING PCSK9 AND USES THEREOF

#1002
20240271142
2024-08-15

COMPOSITIONS AND METHODS FOR THE INHIBITION OF NERVE GROWTH FACTOR AND THE TREATMENT/PREVENTION OF ATRIAL FIBRILLATION

#1003
20240271141
2024-08-15

COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF HEPATITIS B VIRUS (HBV)PROTEIN

#1004
20240271138
2024-08-15

METHODS AND COMPOSITIONS FOR MODULATING STING SIGNALING AND INNATE IMMUNE RESPONSES

#1005
20240271137
2024-08-15

Asymmetric Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof

#1006
20240271136
2024-08-15

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1007
20240271133
2024-08-15

KRAB-Containing Zinc Finger Protein And Cancer

#1008
20240271097
2024-08-15

METHODS AND COMPOSITIONS FOR CELL REPROGRAMMING

#1009
20240269327
2024-08-15

COMPOSITIONS AND METHODS FOR TRANSGENE EXPRESSION

#1010
20240269302
2024-08-15

NANOPARTICLE COMPRISING PEPTIDE-LIPID CONJUGATE FOR DELIVERING OLIGONUCLEOTIDE INTO TARGET CELL AND PHARMACEUTICAL COMPOSITION COMPRISING SAME

#1011
20240269142
2024-08-15

COMBINATION OF A TLR8 MODULATING COMPOUND AND ANTI-HBV siRNA THERAPEUTICS

#1012
20240263175
2024-08-08

COMPOSITION FOR TREATING METASTATIC SOLID CANCER, COMPRISING TSG6 INHIBITOR

#1013
20240261223
2024-08-08

MODULAR LIPID COMPOUNDS AND TWO- TO THREE-COMPONENT LIPID NANOPARTICLE COMPOSITIONS

#1014
20240255880
2024-08-01

SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT

#1015
20240254540
2024-08-01

Methods and Compositions for Determining pH

#1016
20240254493
2024-08-01

COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION

#1017
20240254491
2024-08-01

BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1018
20240254490
2024-08-01

Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof

#1019
20240254489
2024-08-01

COMPOSITIONS AND METHODS OF TARGETING THE PAX6 SIGNALING PATHWAY TO REDUCE FORMATION OF AMYLOID BETA PLAQUES AND NEUROFIBRILLARY TANGLES

#1020
20240254487
2024-08-01

MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1021
20240254486
2024-08-01

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#1022
20240254485
2024-08-01

SIRNAS TARGETING SLC10A1 TRANSCRIPTS, COMPOSITIONS AND USES THEREOF

#1023
20240254482
2024-08-01

METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)

#1024
20240254174
2024-08-01

RABIES VIRAL GLYCOPROTEIN COMPOSITIONS AND METHODS OF USE

#1025
20240252615
2024-08-01

PRE-IMMUNIZATION AND IMMUNOTHERAPY

#1026
20240252600
2024-08-01

COMPOSITIONS AND METHODS FOR PROMOTING THE MINERALIZATION OF BIOLOGICAL TISSUE

#1027
20240247274
2024-07-25

FATTY ACID CONJUGATES OF NUCLEIC ACIDS

#1028
20240247271
2024-07-25

RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)

#1029
20240247267
2024-07-25

Treatment Of Stroke With 1,4-Alpha-Glucan-Branching Enzyme (GBE1) Inhibitors

#1030
20240247266
2024-07-25

METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER

#1031
20240247025
2024-07-25

POLYNUCLEOTIDE CONSTRUCTS

#1032
20240246898
2024-07-25

CATIONIC LIPIDS FOR NUCLEIC ACID DELIVERY AND PREPARATION THEREOF

#1033
20240245784
2024-07-25

TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS

#1034
20240245664
2024-07-25

METHODS OF USING USP15 INHIBITORS

#1035
20240245620
2024-07-25

COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS

#1036
20240240190
2024-07-18

INHIBITORS OF MITOFERRIN-2 FOR USE IN TREATING CANCER

#1037
20240240185
2024-07-18

HOST FACTORS THAT ENHANCE VIRAL PRODUCTION VIA VIRALLY DRIVEN FITNESS-BASED CRISPR SCREENING

#1038
20240240182
2024-07-18

HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1039
20240240178
2024-07-18

SIRNA CONSTRUCTS FOR INHIBITING GENE EXPRESSION IN TARGETED CANCER CELLS

#1040
20240240177
2024-07-18

MULTITARGETING RNA COMPOSITIONS

#1041
20240240176
2024-07-18

PREVENTION OR TREATMENT OF MYOPATHY USING MIR-33B INHIBITOR

#1042
20240238435
2024-07-18

Muscle targeting complexes and uses thereof for treating myotonic dystrophy

#1043
20240238406
2024-07-18

HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY

#1044
20240238027
2024-07-18

IN-SITU CRYO-IMMUNE ENGINEERING FOR CANCER IMMUNOTHERAPY

#1045
20240230644
2024-07-11

METHODS OF TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS

#1046
20240229043
2024-07-11

Methods and Compositions for Treating, Ameliorating, and/or Preventing Chronic Kidney Disease (CKD) and Complications thereof by Regulating DPEP1, CASP9, ACSS2 and/or FASN

#1047
20240229039
2024-07-11

ALLELE-SPECIFIC SILENCING THERAPY FOR DYNAMIN 2-RELATED DISEASES

#1048
20240229034
2024-07-11

LIPID NANOPARTICLES AND METHODS OF USE

#1049
20240229033
2024-07-11

Compositions for Inhibiting Growth of Targeted Cells

#1050
20240229032
2024-07-11

Multitargeting RNA Immunotherapy Compositions

#1051
20240229029
2024-07-11

COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA

#1052
20240229027
2024-07-11

NUCLEIC ACID DELIVERY SYSTEM AND APPLICATION THEREOF

#1053
20240229026
2024-07-11

CHIRAL CONTROL

#1054
20240229025
2024-07-11

siRNA AND USE THEREOF

#1055
20240228660
2024-07-11

VON WILLEBRAND FACTOR (VWF) INHIBITORS

#1056
20240228582
2024-07-11

TM4SF19 INHIBITOR AND USES THEREOF

#1057
20240226331
2024-07-11

METHODS AND COMPOSITIONS FOR REDUCING NUCLEIC ACID VECTOR-INDUCED TOXICITY IN THE INNER EAR

#1058
20240226111
2024-07-11

COMPOSITION FOR TREATING OSTEOARTHRITIS

#1059
20240218371
2024-07-04

METHOD OF TREATING BREAST CANCER IN A SUBJECT BY INHIBITING TUBB2B

#1060
20240218369
2024-07-04

COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS

#1061
20240218368
2024-07-04

COLON CANCER-SPECIFIC TARGET EXOSOME COMPOSITION AS DRUG DELIVERY MATERIAL, AND USE THEREOF

#1062
20240218362
2024-07-04

REPROGRAMMING OF NON-NEURONAL CELLS INTO NEURONS AND METHODS AND COMPOSITIONS TO TREAT NEURODEGENERATIVE DISEASES AND DISORDERS

#1063
20240216531
2024-07-04

CHITOSAN-CONTAINING NANOPARTICLES FOR DELIVERY OF POLYNUCLEOTIDES

#1064
20240216515
2024-07-04

COMPOSITIONS AND METHODS FOR TARGETED DELIVERY TO CELLS

#1065
20240216466
2024-07-04

COMPOSITIONS FOR TREATING HEART DISEASE BY INHIBITING THE ACTION OF mAKAP-beta

#1066
20240216416
2024-07-04

METHOD OF TREATING BREAST CANCER IN A SUBJECT BY INHIBITING TUBB2B

#1067
20240216388
2024-07-04

INHIBITOR OF SUV39H1 HISTONE METHYLTRANSFERASE FOR USE IN CANCER COMBINATION THERAPY

#1068
20240216365
2024-07-04

METHODS AND USES OF PROTEIN DISULFIDE ISOMERASE INHIBITORY COMPOUNDS

#1069
20240209374
2024-06-27

iRNA COMPOSITIONS AND METHODS FOR SILENCING CHITINASE 3-LIKE PROTEIN 1/YKL-40 (CHI3L1/YKL-40) PROTEIN

#1070
20240209373
2024-06-27

ELONGATION OF VERY LONG CHAIN FATTY ACIDS PROTEIN 1 (ELOVL1) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1071
20240209370
2024-06-27

METHODS OF MODULATING ALK

#1072
20240209367
2024-06-27

INHIBITORY NUCLEIC ACIDS FOR FACTOR H FAMILY PROTEINS

#1073
20240209357
2024-06-27

DNA CONSTRUCTS COMPRISING ALTERNATIVE PROMOTERS

#1074
20240209038
2024-06-27

TARGETING PIEZO1 TO TREAT INHERITED AND AGE-RELATED MACULAR DEGENERATIONS

#1075
20240207409
2024-06-27

ORAL DELIVERY OF OLIGONUCLEOTIDES

#1076
20240203526
2024-06-20

SUBSTRATE SEQUENCE DESIGN WORKFLOW FOR THE RNAI-MEDIATED MULTI-SITE REGULATION OF GENOMIC AND SUB-GENOMIC VIRAL RNAS

#1077
20240201194
2024-06-20

METHODS OF DETECTING AND REDUCING CANCER CELL CENTRAL NERVOUS SYSTEM COLONIZATION

#1078
20240201172
2024-06-20

USE OF ODORANT RECEPTOR FOR SUPPRESSING LACTATE-INDUCED M2-TYPE DIFFERENTIATION OF TUMOR-ASSOCIATED MACROPHAGES AND TUMOR GROWTH

#1079
20240200081
2024-06-20

NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE

#1080
20240200080
2024-06-20

DIAGNOSTIC DEVICE FOR LOCAL INTRAVENOUS BIOMARKER MEASUREMENTS AND METHODS OF USE THEREOF

#1081
20240200079
2024-06-20

Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors

#1082
20240200077
2024-06-20

STEAROYL-COA DESATURASE 5 (SCD5) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1083
20240200076
2024-06-20

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#1084
20240200075
2024-06-20

ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1085
20240200074
2024-06-20

METHOD AND COMPOSITIONS FOR PREVENTING TUMOR DEVELOPMENT AND METASTASIS

#1086
20240200063
2024-06-20

MICROGLIAL GENE SILENCING USING DOUBLE-STRANDED SIRNA

#1087
20240200061
2024-06-20

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES

#1088
20240200060
2024-06-20

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#1089
20240197636
2024-06-20

TISSUE-SPECIFIC NUCLEIC ACID DELIVERY BY MIXED CATIONIC LIPID PARTICLES

#1090
20240191240
2024-06-13

DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES

#1091
20240191238
2024-06-13

BIOMARKERS OF AGING FOR DETECTION AND TREATMENT OF DISORDERS

#1092
20240191236
2024-06-13

ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1093
20240191232
2024-06-13

COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION

#1094
20240191230
2024-06-13

CONJUGATES OF SIRNA AND ANTISENSE OLIGONUCLEOTIDES (SIRNASO) AND METHODS OF USE IN GENE SILENCING

#1095
20240191227
2024-06-13

Use of CD56 to predict the differentiation potential of muscle stem cells

#1096
20240189612
2024-06-13

METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES

#1097
20240189435
2024-06-13

NOVEL PEPTIDE-OLIGONUCLEOTIDE CONJUGATE AND USE THEREOF

#1098
20240189339
2024-06-13

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#1099
20240182907
2024-06-06

H-1 PV EXPRESSING RNAi EFFECTORS

#1100
20240182905
2024-06-06

TRANSMEMBRANE PROTEASE, SERINE 6 (TMPRSS6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1101
20240182904
2024-06-06

OLIGONUCLEOTIDES TARGETING S6K1

#1102
20240182902
2024-06-06

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1103
20240182896
2024-06-06

VARIANT RNAi

#1104
20240182895
2024-06-06

Non-liposomal systems for nucleic acid delivery

#1105
20240182893
2024-06-06

INHIBITION OF FGR REDUCES FIBROSIS

#1106
20240182892
2024-06-06

DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS

#1107
20240182561
2024-06-06

CALCIUM VOLTAGE-GATED CHANNEL AUXILIARY SUBUNIT GAMMA 1 (CACNG1) BINDING PROTEINS AND CACNG1-MEDIATED DELIVERY TO SKELETAL MUSCLE

#1108
20240180953
2024-06-06

STAUFEN1 AGENTS AND ASSOCIATED METHODS

#1109
20240175035
2024-05-30

COMPOSITIONS AND METHODS FOR TREATING HYPERCHOLESTEROLEMIA

#1110
20240175034
2024-05-30

FN3 DOMAIN-SIRNA CONJUGATES AND USES THEREOF

#1111
20240175032
2024-05-30

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PCSK9

#1112
20240175031
2024-05-30

TREATMENT OF MST1 RELATED DISEASES AND DISORDERS

#1113
20240175030
2024-05-30

ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1114
20240175028
2024-05-30

DOSING OF siRNA COMPOUNDS TO THE CISTERNA MAGNA

#1115
20240175027
2024-05-30

ANTI-C5 ANTIBODY/C5 IRNA CO-FORMULATIONS AND COMBINATION THERAPIES

#1116
20240175024
2024-05-30

DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES

#1117
20240175023
2024-05-30

GalNAc compositions for improving siRNA bioavailability

#1118
20240175022
2024-05-30

RUNX1 Inhibition for Treatment of Proliferative Vitreoretinopathy and Conditions Associated with Epithelial to Mesenchymal Transition

#1119
20240175019
2024-05-30

Skeletal Muscle Delivery Platforms and Methods of Use

#1120
20240175018
2024-05-30

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

#1121
20240175017
2024-05-30

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1122
20240174604
2024-05-30

Cationic sulfonamide amino lipids and amphiphilic zwitterionic amino lipids

#1123
20240173426
2024-05-30

COMPOSITIONS AND METHODS FOR FIBROBLAST GROWTH FACTOR RECEPTOR 3-MEDIATED DELIVERY TO ASTROCYTES

#1124
20240167041
2024-05-23

LOSS OF LIPID KINASE PI5P4K GAMMA RESTRICTS TUMOR GROWTH

#1125
20240167037
2024-05-23

CANCER THERAPY

#1126
20240167035
2024-05-23

RNAi agents for inhibiting expression of complement component C3 (C3), pharmaceutical compositions thereof, and methods of use

#1127
20240167030
2024-05-23

METHODS AND COMPOSITIONS FOR ACCELERATING OLIGODENDROCYTE MATURATION

#1128
20240167022
2024-05-23

TEMPLATE DIRECTED IMMUNOMODULATION FOR CANCER THERAPY

#1129
20240166998
2024-05-23

METHOD FOR PRODUCING HEMATOPOIETIC CELLS FROM STEM CELLS USING VASCULAR ORGANOIDS

#1130
20240166770
2024-05-23

COMPOSITIONS AND METHODS FOR INHIBITION OF CELL-PENETRATING ANTIBODIES

#1131
20240158798
2024-05-16

NON-VIRAL GENE/CARRIER COMPLEX FOR PREVENTION OR TREATMENT OF ACUTE INFLAMMATORY DISEASE

#1132
20240158796
2024-05-16

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1133
20240158794
2024-05-16

NUCLEOSIDE CONTAINING siRNAS FOR TREATING VIRAL DISEASES

#1134
20240158791
2024-05-16

METHOD OF TREATING FATTY LIVER DISEASE

#1135
20240158789
2024-05-16

NUCLEIC ACIDS SIMULTANEOUSLY INHIBITING EXPRESSION OF C-MET GENE AND PD-L1 GENE

#1136
20240158788
2024-05-16

METHODS AND COMPOSITIONS USED TO MODIFY CHROMATIN ARCHITECTURE TO REGULATE PHENOTYPE IN AGING AND CANCER

#1137
20240158488
2024-05-16

METHODS OF RESTORING FUNCTIONAL CAPACITY AND LINEAGE COMPOSITION OF AN AGING BLOOD AND VASCULAR SYSTEM

#1138
20240156984
2024-05-16

METHODS OF DELIVERING ANIONIC AGENTS IN VIVO USING NON-VIRAL NANOPARTICLE-BASED DELIVERY SYSTEMS

#1139
20240156966
2024-05-16

A SIRNA DRUG, A PHARMACEUTICAL COMPOSITION, A SIRNA-SMALL MOLECULE DRUG CONJUGATE, AND THE APPLICATION THEREOF

#1140
20240150769
2024-05-09

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1141
20240150768
2024-05-09

METHODS FOR THE TREATMENT OF NASH WITH ADVANCED FIBROSIS AND/OR CIRRHOSIS

#1142
20240150767
2024-05-09

SUPEROXIDE DISMUTASE 1 (SOD1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING SUPEROXIDE DISMUTASE 1- (SOD1-) ASSOCIATED NEURODEGENERATIVE DISEASES

#1143
20240150766
2024-05-09

MULTI-CONJUGATE OF SIRNA AND PREPARING METHOD THEREOF

#1144
20240150755
2024-05-09

MODULATING REGULATORY T CELL FUNCTION IN AUTOIMMUNE DISEASE AND CANCER

#1145
20240148875
2024-05-09

Lipid formulations for delivery of therapeutic agents

#1146
20240148835
2024-05-09

TREATING DISORDERS ASSOCIATED WITH DYRK1A DYSFUNCTION

#1147
20240148773
2024-05-09

PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1148
20240148666
2024-05-09

Compositions and methods for organ specific delivery of nucleic acids

#1149
20240141380
2024-05-02

VIRAL VECTOR-BASED RNA DELIVERY SYSTEM AND USE THEREOF

#1150
20240141361
2024-05-02

GENE CIRCUIT, RNA DELIVERY SYSTEM AND USE THEREOF

#1151
20240141358
2024-05-02

SOLUTE CARRIER FAMILY MEMBER IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1152
20240141357
2024-05-02

METHODS AND COMPOSITIONS FOR MODULATING PLASMINOGEN

#1153
20240141353
2024-05-02

SIRNAS AGAINST KRAS AND RAF1

#1154
20240141352
2024-05-02

CHAPERONIN-CONTAINING TCP-1 INHIBITORS FOR THE TREATMENT OF CANCER

#1155
20240141351
2024-05-02

ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE

#1156
20240141348
2024-05-02

ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT

#1157
20240141347
2024-05-02

RNA DELIVERY SYSTEM FOR TREATMENT OF HUNTINGTON'S DISEASE

#1158
20240141345
2024-05-02

CD70-TARGETED MICELLES ENHANCE HIF2? siRNA DELIVERY AND INHIBIT ONCOGENIC FUNCTIONS IN PATIENT-DERIVED CLEAR CELL RENAL CARCINOMA CELLS

#1159
20240141344
2024-05-02

RNA PLASMID DELIVERY SYSTEM AND APPLICATION THEREOF

#1160
20240141337
2024-05-02

RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE

#1161
20240141305
2024-05-02

HSD17B13 VARIANTS AND USES THEREOF

#1162
20240141292
2024-05-02

MODIFICATION OF IMMUNE CELLS FOR REDUCING TOXICITY AND USES THEREOF IN ADOPTIVE CELL THERAPY

#1163
20240138418
2024-05-02

METHODS AND COMPOSITIONS FOR CONTROL OF ARTHROPOD PESTS

#1164
20240132935
2024-04-25

TREATMENT AND DIAGNOSIS OF IMMUNE DISORDERS

#1165
20240132896
2024-04-25

Factor XII (F12) iRNA compositions and methods of use thereof

#1166
20240132895
2024-04-25

GLYCOGEN SYNTHASE KINASE 3 ALPHA (GSK3 ALPHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1167
20240132894
2024-04-25

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

#1168
20240132889
2024-04-25

COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA

#1169
20240132888
2024-04-25

MODIFIED OLIGONUCLEOTIDES TARGETING SNPs

#1170
20240132885
2024-04-25

MODULATION OF TRANSTHYRETIN EXPRESSION

#1171
20240132571
2024-04-25

TM4SF19 INHIBITOR AND USES THEREOF

#1172
20240132554
2024-04-25

METHOD OF TREATMENT OF MALARIA BY TARGETTING OPEN READING FRAMES

#1173
20240131190
2024-04-25

METHODS AND COMPOSITIONS FOR REDUCING NUCLEIC ACID VECTOR-INDUCED TOXICITY IN THE INNER EAR

#1174
20240131174
2024-04-25

PEPTIDIC BLOCKS FOR NUCLEIC ACID DELIVERY

#1175
20240131170
2024-04-25

CATIONIC AMPHIPHILIC POLYMERS FOR CODELIVERY OF HYDROPHOBIC AGENTS AND NUCLEIC ACIDS

#1176
20240124882
2024-04-18

PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1177
20240124880
2024-04-18

Diagnostic kit for metastasis and invasion of breast cancer and use of shRNA molecule for silencing expression of human LINC01614

#1178
20240124879
2024-04-18

RNAI AGENT FOR INHIBITING HBV EXPRESSION AND USE THEREOF

#1179
20240124877
2024-04-18

RNA CLEAVAGE-INDUCED TRANSCRIPT STABILIZER AND USES THEREOF

#1180
20240124876
2024-04-18

COMPOUNDS FOR TREATMENT OF OSTEOARTHRITIS

#1181
20240117362
2024-04-11

Lipid-pegylated compounds, preparations and uses thereof

#1182
20240117361
2024-04-11

COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF GENES

#1183
20240117358
2024-04-11

METHODS AND COMPOSITIONS FOR DIAGNOSING AND TREATING PROSTATE CANCER BASED ON LONG NONCODING RNA OVERLAPPING THE LCK GENE THAT REGULATES PROSTATE CANCER CELL GROWTH

#1184
20240117355
2024-04-11

LIPOPROTEIN-MIMICKING SOLID LIPID NANOPARTICLES FOR DRUG DELIVERY AND USES THEREOF

#1185
20240117354
2024-04-11

COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF GENES

#1186
20240117349
2024-04-11

iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)

#1187
20240116973
2024-04-11

MODIFIED OLIGONUCLEOTIDES

#1188
20240115679
2024-04-11

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#1189
20240115556
2024-04-11

A JMJD6 TARGETING AGENT FOR TREATING PROSTATE CANCER

#1190
20240110202
2024-04-04

Advanced Cell-Permeable Peptide Carriers

#1191
20240110188
2024-04-04

PREVENTION AND/OR TREATMENT OF INFLAMMATORY SKIN DISEASE

#1192
20240110187
2024-04-04

METHODS FOR PROPHYLACTIC AND THERAPEUTIC TREATMENT OF 2019-nCoV USING siRNAs AGAINST ORF1AB and N-Protein

#1193
20240110180
2024-04-04

COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES

#1194
20240109931
2024-04-04

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

#1195
20240108741
2024-04-04

COMBINATION siRNA AND PEPTIDE DOCKING VEHICLE (PDoV) COMPOSITIONS AND METHODS OF THEIR USE FOR IMPROVED REGULATION AND FUNCTIONALITY

#1196
20240108734
2024-04-04

METHODS FOR TREATING AND AMELIORATING CANCER

#1197
20240108714
2024-04-04

PRE-IMMUNIZATION AND IMMUNOTHERAPY

#1198
20240102107
2024-03-28

METHODS AND COMPOSITIONS RELATED TO T-CELL ACTIVITY

#1199
20240102019
2024-03-28

COMPOSITION COMPRISING EMP3 INHIBITOR FOR INHIBITING GROWTH OF CANCER STEMCELL AND USE THEREOF

#1200
20240102017
2024-03-28

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF