109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
COMPOSITIONS AND METHODS FOR TREATMENT OF PAIN
#602TARGETED EXTRACELLULAR VESICLES FOR DELIVERY OF THERAPEUTICS
#603COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#604METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS
#605COMPOSITIONS FOR AQUACULTURING
#606COMPOSITIONS AND METHODS TO TREAT CANCER
#607MEANS AND METHODS FOR REDUCING TUMORIGENICITY OF CANCER STEM CELLS
#608METHODS OF CANCER TREATMENT BY INHIBITION OF VASCULOGENESIS AND GLI1
#609siRNAs and shRNAs Targeting HIV and Combinations, Expression Cassettes, Cells and Use Thereof
#610MODIFICATION PATTERNS FOR SMALL INTERFERING RNA MOLECULES WITH HIGH STABILITY AND GENE SILENCING ACTIVITIES
#611DEAMINASE-BASED RNA SENSORS
#612ADVANCED RNA TARGETING (ARNATAR)
#613METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#614MODIFIED siRNA FOR SELECTIVELY INHIBITING EXPRESSION OF MUTANT FUS
#615METHODS AND COMPOSITIONS FOR CARDIAC MODELS
#616TARGETED COMPOSITIONS
#617CARRIER FOR PROMOTING FENTON REACTION AND PREPARATION PROCESS AND USES THEREOF
#618CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING
#619LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF
#620Method for Regulating and Controlling Heterologous Synthetic Flavonoid Compound and Use Thereof
#621COMPOSITIONS AND METHODS FOR INHIBITING KETOHEXOKINASE (KHK)
#622GENE THERAPY TARGETING THE NEONATAL FORM OF NAV1.5 FOR TREATING CANCER
#623Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors
#624A GLUN2D INHIBITOR FOR USE IN THE TREATMENT OR RELAPSE PREVENTION OF A DEPRESSIVE EPISODE
#625BANCR Compositions and Methods for Treating Disease
#626COMPOSITIONS AND METHODS USEFUL IN PROMOTING MILK PRODUCTION
#627TREATMENT AND PREVENTION OF ALCOHOLIC LIVER DISEASE
#628Trialkyne Linking Agents and Methods of Use
#629Cationic Hyperbranched Starch-based Gene Carrier, Preparation Method and Application Thereof
#630Neurosome/Astrosome Compositions and Methods of Use
#631CANNULA SYSTEM AND USE THEREOF
#632TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#633Treatment Of Acne Rosacea With Pancreatic Lipase-Related Protein 3 (PNLIPRP3) Inhibitors
#634COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#635HEPARIN SULFATE BIOSYNTHESIS PATHWAY ENZYME IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#636TARGETING OF XKR8 IN THERAPIES
#637PHARMACEUTICAL COMPOSITION FOR SUPPRESSING INVASION OF CANCER, AND METHOD FOR SUPPRESSING INVASION OF CANCER
#638COMPOSITIONS AND METHODS FOR TREATING CANCER
#639TREATMENT OF BRAIN TUMORS BY TARGETING THE CHOLESTEROL PATHWAY IN ASTROCYES
#640COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND TARGETED SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS
#641m6A mRNA MODIFICATION IN CANCER TREATMENT
#642Method of Targeting Cells and Associated Compositions
#643HIF1A OR GLUT1 INHIBITION IN INFLAMMATORY SKIN DISEASES
#644Treatment Of Muscle Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors
#645RNAi Agents for Inhibiting Expression of Inhibin Subunit Beta E (INHBE), Pharmaceutical Compositions Thereof, and Methods of Use
#646TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES
#647RNAS FOR COMPLEMENT INHIBITION
#648OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION
#649AGENTS AND METHODS FOR PREVENTING OR INHIBITING ADAPTIVE IMMUNE RESPONSES ASSOCIATED WITH MULTIPLE SCLEROSIS
#650NOVEL CATIONIC LIPID COMPOUNDS
#651HYPERBRANCHED POLY(BETA-AMINO ESTER) FOR SIRNA DELIVERY AND GENE SILENCING
#652SMALL MOLECULE AND SIRNA INHIBITORS AGAINST LIPOCALIN-2
#653PREKALLIKREIN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#654DETECTION OF GENETIC VARIANTS OF THE BETA-ADRENERGIC RECEPTOR PATHWAY FOR DETECTING AND TREATING RETINOPATHY OF PREMATURITY
#655DNA Amplification Method Using CARE Elements
#656Application of PRDX5 and GPX4 Genes in Preparation of Drugs for Castration-resistant Prostate Cancer
#657RNA INTERFERENCE MEDIATED INHIBITION OF PROLYL HYDROXYLASE DOMAIN 2 (PHD2) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#658AGT Inhibitor and Use Thereof
#659USE OF CCL7 ANTAGONISTS FOR THE PREVENTION OR TREATMENT OF DIABETIC KIDNEY DISEASE
#660Composition for Administration of Double-Stranded Oligonucleotide Structures Using Ultrasonic Nebulizer for Prevention or Treatment of Respiratory Viral Infection Including COVID-19, Pulmonary Fibrosis Caused by Viral Infection, or Respiratory Diseases
#661OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING
#662Advanced RNA targeting (ARNATAR) for angiotensinogen
#663METHODS AND MATERIALS FOR TREATING HEART ATTACK
#664COMPOSITIONS AND METHODS FOR TRANSFER USING CER1
#665AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENTS
#666MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF
#667ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#668DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF
#669IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#670COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#671METHODS FOR THE TREATMENT OF NLRP3 RELATED DISORDERS
#672Heterocyclic Carboxylate Compounds as Glycolate Oxidase Inhibitors
#673COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH
#674ENHANCED PRODUCTION OF SQUALENE IN PLANT SYSTEMS
#675METHODS AND COMPOSITIONS FOR TARGETED TRANS-SPLICING
#676CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#677COMPOSITIONS AND METHODS OF tRNA SILENCING
#678TUNABLE REVERSIR TM COMPOUNDS
#679OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#680BIOACTIVE CONJUGATES FOR OLIGONUCLEOTIDE DELIVERY
#681Chimeric Antigen Receptor-T Cells Targeting HIV-Infected Cells
#682NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING NUCLEIC ACID, PREPARATION METHOD THEREFOR AND USE THEREOF
#683COMPOSITIONS FOR RNA-PROTEIN TETHERING AND METHODS OF USING
#684METHODS AND COMPOSITIONS RELATED TO RNA-TARGETED RHO SMALL GTPase RND3/RhoE THERAPY
#685DIRECT PRODUCTION OF SIRNAS IN SACCHAROMYCES BOULARDII AND PACKAGING IN EXTRACELLULAR VESICLES (EVs) FOR TARGETED GENE SILENCING
#686MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF
#687iRNA Compositions and Methods for Silencing MYLIP
#688APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#689CELLS COMPRISING A SUPPRESSOR OF GENE EXPRESSION AND/OR A SYNTHETICPATHWAY ACTIVATOR AND/OR AN INDUCIBLE PAYLOAD
#690TRANSMISSIBLE ELEMENTS COMPRISING PATHWAY MODIFICATION SYSTEMS AND EXOGENOUS NUCLEIC ACIDS FOR THE PRODUCTION OF MOLECULES OF INTEREST
#6913-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#692PRODUCTS AND COMPOSITIONS
#693METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#694ATTENUATED ORTHOMYXOVIRUS-BASED VECTOR PLATFORM
#695TREATMENT OF FGG RELATED DISEASES AND DISORDERS
#696SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#697GENETICALLY MODIFIED BIOPROSTHETIC HEART VALVE AND PRODUCTION METHOD THEREOF
#698EXTRACTION OF PLANT SOURCE "MEDICINAL SOUP" AND MANUAL PREPARATION OF "HERBAL MEDICINE" AND RELATED PRODUCTS
#699Subcutaneous Delivery of RNAi Agents for Inhibiting Expression of Receptor for Advanced Glycation End-products
#700RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Compositions Thereof, and Methods of Use
#701Double Stranded Oligonucleotide For Modulating JAK1 Expression
#702OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS
#703CIRCULAR RNA DERIVED FROM RNA VIRUSES AND RELATED COMPOSITIONS AND METHODS
#704MODIFIED DOUBLE-STRANDED RNA AGENTS
#705NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
#706STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#707CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#708COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#709GLYCAN CONJUGATE COMPOSITIONS AND METHODS
#710Novel Compositions for Conjugating Oligonucleotides and Carbohydrates
#711COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#712TEMPERATURE-BASED TRANSIENT DELIVERY OF NUCLEIC ACIDS AND PROTEINS TO CELLS AND TISSUES
#713COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY
#714USE OF MfERF026 GENE REGULATION IN GROWTH, DEVELOPMENT, AND STRESS TOLERANCE OF MEDICAGO SATIVA
#715LIPID-PEGYLATED COMPOUNDS, PREPARATIONS AND USES THEREOF
#716COMPOSITIONS AND METHODS FOR TREATMENT OF CANCERS USING MODIFIED siRNA-GEM AGENTS
#717COMPOSITIONS AND METHODS FOR TREATING ALZHEIMER'S DISEASE UTILIZING A TRANSCRIPTIONAL MASTER REGULATOR OF THE RETROMER COMPLEX
#718STAGGERED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS
#719Compositions And Methods For Differentiation Of Human Pluripotent Stem Cells Into Desired Cell Types
#720MUSCLE TARGETING COMPLEXES FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#721NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF TMPRSS6 AND IRON CHELATORS
#722METHODS OF TARGETING RNF213 SIGNALING PATHWAY FOR TREATING DISEASES
#723HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS
#724NOVEL OXO-RNA COMPOSITIONS AND THE RELATED APPLICATIONS THEREOF
#725METHODS FOR THE TREATMENT OF HRD CANCER AND BRCA-ASSOCIATED CANCER
#726PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING TARGET CANCER INCLUDING BRCA-SPECIFIC siRNA AS ACTIVE INGREDIENT
#727COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#728IRNA COMPOSITIONS AND METHODS FOR SILENCING COMPLEMENT COMPONENT 3 (C3)
#729TARGETING LIGAND AND USE THEREOF
#730ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV)
#731LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY
#732PHARMACEUTICAL COMPOSITION FOR PROMOTING CANCER IMMUNOTHERAPY AND METHOD FOR PROMOTING CANCER IMMUNOTHERAPY
#733AGENTS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS
#734Methods for the Modification of Cells, Modified Cells and Uses Thereof
#735IRAP INHIBITORS FOR USE IN THE TREATMENT OF INFLAMMATORY DISEASES
#736Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#737NUCLEIC ACID INTERFERENCE PHARMACEUTICAL COMPOSITION, AND DRUG FOR TREATING COLORECTAL CANCER, GASTRIC CANCER, AND PROSTATE CANCER
#738COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS
#739APP iRNA Compositions and Methods of Use Thereof for Treating or Preventing Diseases Characterized by Enlarged Endosomes
#740HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#741PROBES FOR DEPLETING ABUNDANT SMALL NONCODING RNA
#742TARGETING APOE ENHANCES T-CELL KILLING IN CANCER IMMUNOTHERAPY
#743PEPTIDE-BINDING HYBRID LIPOSOME EXOSOME, PEPTIDE-BINDING EXOSOME, COMPOSITION CONTAINING SAME, AND METHOD OF FORMING SAME
#744COMPOSITIONS AND METHODS OF ALLEVIATING RESISTANCE TO CHEMOTHERAPY
#745METHODS AND COMPOSITIONS FOR TARGETING ALTERNATIVE METABOLISM ALONG WITH FLT3 INHIBITOR-MEDIATED ANTILEUKEMIC ACTIONS
#746PHOTO-CROSSLINKED BIOREDUCIBLE POLYMERIC NANOPARTICLES FOR ENHANCED RNA DELIVERY
#747METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESISTANT INFLAMMATORY DISEASES
#748GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS
#749COMPOSITIONS AND METHODS FOR TREATMENT OF MIC60 DEPLETED CANCERS AND METASTASIS
#750COMPOSITION FOR DIAGNOSIS, PREVENTION, OR TREATMENT OF VASCULAR SMOOTH MUSCLE CELL PROLIFERATIVE DISEASE, USING MIRNA INHIBITOR
#751NUCLEIC ACIDS CONTAINING ABASIC NUCLEOSIDES
#752TREATMENT OF COMPLEMENT-MEDIATED DISORDERS
#753COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT COMPONENT 3 EXPRESSION
#754Composition for inducing direct reprogramming comprising self-assembled RNA construct
#755Glioblastoma Multiforme Treatments
#756BLOCK COPOLYMERS AND USES THEREOF
#757Lipid nanoparticle compositions and uses thereof
#758POLY-GA PROTEINS IN ALZHEIMER’S DISEASE
#759ANTISENSE OLIGONUCLEOTIDES HAVING ONE OR MORE ABASIC UNITS
#760USE OF PI3KC2B INHIBITORS FOR THE PRESERVATION OF VASCULAR ENDOTHELIAL CELL BARRIER INTEGRITY
#761SIRNA STRUCTURES FOR HIGH ACTIVITY AND REDUCED OFF TARGET
#762OLIGONUCLEOTIDES FOR SARS-CoV-2 MODULATION
#763PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV
#764Means and Methods for Chronic Wound Healing
#765Compositions and Methods for Treating Cag Repeat Diseases
#766KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#767MODIFIED SMALL INTERFERING RNA MOLECULES WITH REDUCED OFF-TARGET EFFECTS
#768Compositions For and Methods of Improving Viral Vectors
#769PEPTIDE HAVING INDEPENDENTLY STABILIZED HYDROPHOBIC ALPHA HELIX, PEPTIDE COMPLEX COMPRISING SAME AND USES THEREOF
#770TARGETING NANOPARTICLES FOR THERAPY
#771NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#772METHODS AND COMPOSITIONS FOR TARGETING SV2 PROTEINS FOR IMMUNE REGULATION
#773Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#774ORAL CODELIVERY OF 5-FLUOREURACIL AND Bcl2 siRNA TREATING STOMACH CANCER
#775AN ANTI-INFLAMMATORY COMPOSITION AND A METHOD OF OBTAINING THE SAME
#776OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION
#777METHODS AND COMPOSITIONS FOR PROMOTING SURVIVAL & PROLIFERATION OF ENDOTHELIAL CELLS & STIMULATING ANGIOGENESIS
#778ORAL THERAPEUTIC VACCINE COMPOSITIONS, METHODS AND TREATMENT OF COVID
#779COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#780ORAL CODELIVERY OF NAVITOCLAX AND Bcl2 siRNA TREATING GASTIC CANCER
#781RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S SYNDROME
#782COMPOSITIONS AND METHODS FOR THE INHIBITION OF TUMOR METASTASIS AND HORIZONTAL GENE TRANSFER
#783iRNA Compositions and Methods for Targeting ANGPTL7
#784MODIFIED DOUBLE-STRANDED RNA AGENTS
#785LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF CENTRAL NERVOUS SYSTEM DISEASES
#786RNAi TARGETING HNRNPH2 MISSENSE MUTATIONS FOR TREATMENT OF BAIN SYNDROME
#787RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSOCIATED NEUROLOGICAL DISORDER
#788Atg8ylation coordinates stress granule formation and mTOR inactivation in response to lysosomal damage
#789FOXO1-TARGETED THERAPY FOR THE TREATMENT OF CANCER
#790CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TREATING NEUROLOGICAL DISEASES
#791POLYCATIONIC METHYL PHOSPHOLIPIDS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS
#792Muscle targeting complexes and uses thereof for treating dystrophinopathies
#793CELL-DERIVED NANOVESICLES FOR IN VIVO TRANSPORT AND DELIVERY OF THERAPEUTIC MATERIALS
#794COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION
#795COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#796METHOD OF REGULATING PULMONARY ARTERY VASCULAR REMODELING
#797ADAMTS14 INHIBITION
#798FACTOR XII (F12) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#799INHIBITION OF NEUROFIBRILLARY TANGLES USING OLIGONUCLEOTIDES AGAINST CIRCULAR RNAS FROM THE MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) LOCUS
#800Compositions and methods for inhibiting LPA expression
#801ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#802TUMOR DELIVERY OF DENDRITIC OLIGONUCLEOTIDES
#803IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#804Compounds and Methods for Reducing ATXN2 Expression
#805AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#806SGF29 AS A TARGET FOR HOX/MYC DRIVEN CANCERS
#807Muscle targeting complexes and uses thereof for treating dystrophinopathies
#808METHODS OF TREATING CANCER HAVING AN ACTIVE WNT/BETA-CATENIN PATHWAY
#809COMPOSITIONS AND METHODS FOR GENERATING SYNTHETIC LETHALITY IN TUMORS
#810CATIONIC POLYMERS
#811METHODS FOR ALTERING GENE EXPRESSION FOR GENETIC DISORDERS
#812TREATMENT OF MST1R RELATED DISEASES AND DISORDERS
#813Treatment of MST1 related diseases and disorders
#814TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#815RNAi Agents for Inhibiting Expression of Coronavirus (CoV) Viral Genomes, Compositions Thereof, and Methods of Use
#816LIGAND CONJUGATES FOR DELIVERY OF THERAPEUTICALLY ACTIVE AGENTS
#817Site-Specific Crosslinking of Antibodies
#818NKD2 AS TARGET FOR TREATING RENAL FIBROSIS
#819IONIZABLE CATIONIC LIPIDS FOR RNA DELIVERY
#820Gene-regulating compositions and methods for improved immunotherapy
#821INHIBITOR OLIGONUCLEOTIDES AND METHODS OF USE THEREOF
#822COMPOSITIONS FOR AND METHODS OF TREATING AND/OR PREVENTING GLUTARIC ACIDURIA TYPE-1
#823HSD17B13-RELATED DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#824TARGETED GENE THERAPY FOR DM-1 MYOTONIC DYSTROPHY
#825Method For Promoting Differentiation Of Pluripotent Stem Cells By Reducing Undifferentiated State Thereof
#826MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#827CONJUGATED OLIGONUCLEOTIDES AND USES THEREOF
#828MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR MODULATION OF GENES ASSOCIATED WITH MUSCLE HEALTH
#829RNA binding and stabilising cationic liposome, its application and method of loading the liposome with emetine
#830LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#831PLANT VECTORS, COMPOSITIONS AND USES RELATING THERETO
#832COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#833NUCLEIC ACID TARGETING PROPROTEIN CONVERTASE SUBTILISIN/KEXIN 9 AND USES THEREOF
#834COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF ANGIOPOIETIN-LIKE 3 (ANGPTL3) PROTEIN
#835Treatment of Liver Diseases With Cell Death Inducing DFFA Like Effector B (CIDEB) Inhibitors
#836ENGINEERED PRODUCER CELL LINES AND METHODS OF MAKING AND USING THE SAME
#837TKTL1 INHIBITORS FOR ANTIVIRAL THERAPY
#838INCLUSION BODY MEDIATED METHOD FOR DOUBLE-STRANDED RNA PRODUCING
#839IL-34 ANTISENSE AGENTS AND METHODS OF USING SAME
#840NCOVSIRNA DRUG FOR TARGETED DELIVERY SHRNA by RBD, SYNTHESIS METHOD, AND APPLICATION THEREOF
#841NOVEL COMPOUND AND APPLICATION THEREOF
#842PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING CANCER, CONTAINING CD300C EXPRESSION INHIBITOR OR ACTIVITY INHIBITOR
#843HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#844Targeting GPR65 for the Treatment of Cancer in Overweight and Obese Individuals
#845ACTIVATION OF SURVIVIN-SPECIFIC IMMUNE RESPONSES USING DENDRITIC CELL DERIVED EXOSOMES
#846METHODS FOR THE TREATMENT OF OCULAR ROSACEA
#847SELECTIVE INHIBITORS OF ROCK2 FOR THE TREATMENT OF MUSCULAR DYSTROPHY
#848SELF-INACTIVATING VECTORS FOR GENE EDITING
#849SYNTHETIC RNAS AND USES THEREOF
#850RENAL INJURY BIOMARKERS AS BIOMARKERS FOR ACUTE HEPATIC PORPHYRIA (AHP)
#851LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#852CANCER TREATMENT USING siRNA TO MODULATE EXPRESSION OF PRDM2/RIZ PROTEIN
#853DENDRITIC CONJUGATES FOR THE BRAIN DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#854TREATMENT OF FIBROSIS
#855MULTIGENE CONSTRUCTS FOR TREATMENT OF AGE-RELATED MACULAR DEGENERATION AND OTHER COMPLEMENT DYSREGULATION-RELATED CONDITIONS
#856EXTRAHEPATIC DELIVERY
#857GASDERMIN-D INHIBITORS AND USES THEREOF FOR TREATING PULMONARY VASO-OCCLUSION
#858High Efficiency Beef Cattle Having Modified ACTN3 Genes
#859HAIRPIN NUCLEIC ACID COMPOSITION
#860Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#861SNRNA TARGETING USH2A PRE-MRNA AND APPLICATION THEREOF
#862COMPOSITIONS AND METHODS FOR SIRNA TREATMENT OF MUSCULAR DYSTROPHY
#863DOUBLE STRANDED NUCLEIC ACID COMPOUNDS INHIBITING ZPI
#864CONTROL OF INSECT INFESTATION
#865THREE-DIMENSIONAL DIRECT NEURONAL REPROGRAMMING TO MODEL ALZHEIMER'S DISEASE IN HUMAN NEURONS
#866COSTIMULATORY B7-H1 IN RENAL CELL CARCINOMA PATIENTS: INDICATOR OF TUMOR AGGRESSIVENESS AND POTENTIAL THERAPEUTIC TARGET
#867PHARMACEUTICAL COMPOSITIONS TARGETING IMMUNE-MEDIATED PROCESSES IN NEURODEGENERATIVE DISEASE
#868INHIBITION OF KYNURENINE SYNTHESIS AND/OR SIGNALING TO TREAT LEUKEMIA AND MYELODYSPLASIA
#869METHODS FOR TREATMENT OF NEURON DEGENERATION
#870METHODS FOR MODULATING THE REGENERATIVE PHENOTYPE IN MAMMALIAN CELLS
#871DENDRITIC CONJUGATES FOR THE SKIN DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#872PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#873TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS
#874Products and Methods for Treatment of Amyotrophic Lateral Sclerosis
#875METHODS AND COMPOSITIONS FOR TREATING SUBJECTS HAVING OR AT RISK OF DEVELOPING A NON-PRIMARY HYPEROXALURIA DISEASE OR DISORDER
#876DUAL FUNCTION HYBRID NANOPARTICLES AND METHODS OF USING THE SAME TO TREAT DISEASES AND DISORDERS
#877COMPOSITIONS AND METHODS FOR INHIBITING LPA EXPRESSION
#878SPINK1 AS A TARGET FOR THERAPEUTIC INTERVENTION IN LUNG DISEASES
#879METHODS FOR TREATING SICKLE CELL DISEASE OR BETA THALASSEMIA USING COMPLEMENT ALTERNATIVE PATHWAY INHIBITORS
#880A SHORTENED P63-PROTEIN DOMAIN TO ENHANCE HUMAN CARDIAC REPROGRAMMING
#881TREATMENT OF CANCERS OR NEOPLASMS BY INHIBITING KIF15
#882CATIONIC LIPID, LIPOSOME CONTAINING CATIONIC LIPID, AND NUCLEIC-ACID PHARMACEUTICAL COMPOSITION CONTAINING LIPOSOME AND FORMULATION AND APPLICATION THEREOF
#883INHIBITORS OF EXPRESSION AND/OR FUNCTION
#884USE OF OLIGONUCLEOTIDES FOR INDIVIDUALS WITH RENAL IMPAIRMENT
#885METHODS OF CONTROLLING RNA BINDING PROTEIN ACTIVITY
#886COMPOSITIONS AND METHODS FOR INHIBITING THE EXPRESSION OF TMIGD2
#887COMPOUNDS AND METHODS FOR REDUCING DUX4 EXPRESSION
#8882'-MODIFIED NUCLEOSIDE BASED OLIGONUCLEOTIDE PRODRUGS
#889PRODUCTS AND METHODS FOR PROMOTING MYOGENESIS
#890A NON-CANONICAL SIGNALING ACTIVITY OF CGAMP TRIGGERS DNA DAMAGE RESPONSE SIGNALING
#891ANTISENSE OLIGONUCLEOTIDES TARGETING UNC13A
#892NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#893GALNAC-MONOMERS AND GALNAC-NUCLEIC ACID CONJUGATES
#894COMPOSITIONS COMPRISING DOPED SILICON PARTICLES, AND RELATED METHODS
#895NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF
#896MODULATORS OF ENaC EXPRESSION
#897MODIFIED OLIGONUCLEOTIDES TARGETING SNPs
#898METHODS FOR REACTIVATING GENES ON THE INACTIVE X CHROMOSOME
#899LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE
#900NUCLEIC ACID CONSTRUCT ENABLING EXPRESSION AND INHIBITION OF GENE SIMULTANEOUSLY