ClassID:

109145

C12N2310/14 - page 3 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.

Recent Application in this class:
#601
20250109402
2025-04-03

COMPOSITIONS AND METHODS FOR TREATMENT OF PAIN

#602
20250109400
2025-04-03

TARGETED EXTRACELLULAR VESICLES FOR DELIVERY OF THERAPEUTICS

#603
20250108120
2025-04-03

COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES

#604
20250108111
2025-04-03

METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS

#605
20250108067
2025-04-03

COMPOSITIONS FOR AQUACULTURING

#606
20250101435
2025-03-27

COMPOSITIONS AND METHODS TO TREAT CANCER

#607
20250101433
2025-03-27

MEANS AND METHODS FOR REDUCING TUMORIGENICITY OF CANCER STEM CELLS

#608
20250101430
2025-03-27

METHODS OF CANCER TREATMENT BY INHIBITION OF VASCULOGENESIS AND GLI1

#609
20250101429
2025-03-27

siRNAs and shRNAs Targeting HIV and Combinations, Expression Cassettes, Cells and Use Thereof

#610
20250101428
2025-03-27

MODIFICATION PATTERNS FOR SMALL INTERFERING RNA MOLECULES WITH HIGH STABILITY AND GENE SILENCING ACTIVITIES

#611
20250101426
2025-03-27

DEAMINASE-BASED RNA SENSORS

#612
20250101423
2025-03-27

ADVANCED RNA TARGETING (ARNATAR)

#613
20250101422
2025-03-27

METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT

#614
20250101420
2025-03-27

MODIFIED siRNA FOR SELECTIVELY INHIBITING EXPRESSION OF MUTANT FUS

#615
20250101383
2025-03-27

METHODS AND COMPOSITIONS FOR CARDIAC MODELS

#616
20250099594
2025-03-27

TARGETED COMPOSITIONS

#617
20250099591
2025-03-27

CARRIER FOR PROMOTING FENTON REACTION AND PREPARATION PROCESS AND USES THEREOF

#618
20250099497
2025-03-27

CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING

#619
20250099394
2025-03-27

LIPID NANOPARTICLE COMPOSITIONS AND USES THEREOF

#620
20250092431
2025-03-20

Method for Regulating and Controlling Heterologous Synthetic Flavonoid Compound and Use Thereof

#621
20250092403
2025-03-20

COMPOSITIONS AND METHODS FOR INHIBITING KETOHEXOKINASE (KHK)

#622
20250092399
2025-03-20

GENE THERAPY TARGETING THE NEONATAL FORM OF NAV1.5 FOR TREATING CANCER

#623
20250092396
2025-03-20

Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors

#624
20250092395
2025-03-20

A GLUN2D INHIBITOR FOR USE IN THE TREATMENT OR RELAPSE PREVENTION OF A DEPRESSIVE EPISODE

#625
20250092394
2025-03-20

BANCR Compositions and Methods for Treating Disease

#626
20250092129
2025-03-20

COMPOSITIONS AND METHODS USEFUL IN PROMOTING MILK PRODUCTION

#627
20250092126
2025-03-20

TREATMENT AND PREVENTION OF ALCOHOLIC LIVER DISEASE

#628
20250092072
2025-03-20

Trialkyne Linking Agents and Methods of Use

#629
20250090685
2025-03-20

Cationic Hyperbranched Starch-based Gene Carrier, Preparation Method and Application Thereof

#630
20250090460
2025-03-20

Neurosome/Astrosome Compositions and Methods of Use

#631
20250090197
2025-03-20

CANNULA SYSTEM AND USE THEREOF

#632
20250084435
2025-03-13

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#633
20250084419
2025-03-13

Treatment Of Acne Rosacea With Pancreatic Lipase-Related Protein 3 (PNLIPRP3) Inhibitors

#634
20250084418
2025-03-13

COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION

#635
20250084417
2025-03-13

HEPARIN SULFATE BIOSYNTHESIS PATHWAY ENZYME IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#636
20250084416
2025-03-13

TARGETING OF XKR8 IN THERAPIES

#637
20250084415
2025-03-13

PHARMACEUTICAL COMPOSITION FOR SUPPRESSING INVASION OF CANCER, AND METHOD FOR SUPPRESSING INVASION OF CANCER

#638
20250084148
2025-03-13

COMPOSITIONS AND METHODS FOR TREATING CANCER

#639
20250082766
2025-03-13

TREATMENT OF BRAIN TUMORS BY TARGETING THE CHOLESTEROL PATHWAY IN ASTROCYES

#640
20250082759
2025-03-13

COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND TARGETED SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS

#641
20250082733
2025-03-13

m6A mRNA MODIFICATION IN CANCER TREATMENT

#642
20250082679
2025-03-13

Method of Targeting Cells and Associated Compositions

#643
20250075218
2025-03-06

HIF1A OR GLUT1 INHIBITION IN INFLAMMATORY SKIN DISEASES

#644
20250075216
2025-03-06

Treatment Of Muscle Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors

#645
20250075214
2025-03-06

RNAi Agents for Inhibiting Expression of Inhibin Subunit Beta E (INHBE), Pharmaceutical Compositions Thereof, and Methods of Use

#646
20250075211
2025-03-06

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES

#647
20250075209
2025-03-06

RNAS FOR COMPLEMENT INHIBITION

#648
20250075208
2025-03-06

OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION

#649
20250074966
2025-03-06

AGENTS AND METHODS FOR PREVENTING OR INHIBITING ADAPTIVE IMMUNE RESPONSES ASSOCIATED WITH MULTIPLE SCLEROSIS

#650
20250074867
2025-03-06

NOVEL CATIONIC LIPID COMPOUNDS

#651
20250073342
2025-03-06

HYPERBRANCHED POLY(BETA-AMINO ESTER) FOR SIRNA DELIVERY AND GENE SILENCING

#652
20250073257
2025-03-06

SMALL MOLECULE AND SIRNA INHIBITORS AGAINST LIPOCALIN-2

#653
20250073256
2025-03-06

PREKALLIKREIN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF

#654
20250066855
2025-02-27

DETECTION OF GENETIC VARIANTS OF THE BETA-ADRENERGIC RECEPTOR PATHWAY FOR DETECTING AND TREATING RETINOPATHY OF PREMATURITY

#655
20250066811
2025-02-27

DNA Amplification Method Using CARE Elements

#656
20250066794
2025-02-27

Application of PRDX5 and GPX4 Genes in Preparation of Drugs for Castration-resistant Prostate Cancer

#657
20250066791
2025-02-27

RNA INTERFERENCE MEDIATED INHIBITION OF PROLYL HYDROXYLASE DOMAIN 2 (PHD2) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)

#658
20250066789
2025-02-27

AGT Inhibitor and Use Thereof

#659
20250066788
2025-02-27

USE OF CCL7 ANTAGONISTS FOR THE PREVENTION OR TREATMENT OF DIABETIC KIDNEY DISEASE

#660
20250066787
2025-02-27

Composition for Administration of Double-Stranded Oligonucleotide Structures Using Ultrasonic Nebulizer for Prevention or Treatment of Respiratory Viral Infection Including COVID-19, Pulmonary Fibrosis Caused by Viral Infection, or Respiratory Diseases

#661
20250066780
2025-02-27

OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING

#662
20250066779
2025-02-27

Advanced RNA targeting (ARNATAR) for angiotensinogen

#663
20250066778
2025-02-27

METHODS AND MATERIALS FOR TREATING HEART ATTACK

#664
20250066741
2025-02-27

COMPOSITIONS AND METHODS FOR TRANSFER USING CER1

#665
20250064958
2025-02-27

AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENTS

#666
20250064944
2025-02-27

MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF

#667
20250064943
2025-02-27

ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#668
20250064940
2025-02-27

DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF

#669
20250064938
2025-02-27

IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING

#670
20250064936
2025-02-27

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#671
20250064808
2025-02-27

METHODS FOR THE TREATMENT OF NLRP3 RELATED DISORDERS

#672
20250064787
2025-02-27

Heterocyclic Carboxylate Compounds as Glycolate Oxidase Inhibitors

#673
20250064752
2025-02-27

COMPOSITIONS FOR THE DELIVERY OF tRNA AS NANOPARTICLES AND METHODS OF USE THEREWITH

#674
20250059546
2025-02-20

ENHANCED PRODUCTION OF SQUALENE IN PLANT SYSTEMS

#675
20250059543
2025-02-20

METHODS AND COMPOSITIONS FOR TARGETED TRANS-SPLICING

#676
20250059542
2025-02-20

CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#677
20250059538
2025-02-20

COMPOSITIONS AND METHODS OF tRNA SILENCING

#678
20250059536
2025-02-20

TUNABLE REVERSIR TM COMPOUNDS

#679
20250059535
2025-02-20

OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES

#680
20250059533
2025-02-20

BIOACTIVE CONJUGATES FOR OLIGONUCLEOTIDE DELIVERY

#681
20250057884
2025-02-20

Chimeric Antigen Receptor-T Cells Targeting HIV-Infected Cells

#682
20250057870
2025-02-20

NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING NUCLEIC ACID, PREPARATION METHOD THEREFOR AND USE THEREOF

#683
20250051788
2025-02-13

COMPOSITIONS FOR RNA-PROTEIN TETHERING AND METHODS OF USING

#684
20250051782
2025-02-13

METHODS AND COMPOSITIONS RELATED TO RNA-TARGETED RHO SMALL GTPase RND3/RhoE THERAPY

#685
20250051774
2025-02-13

DIRECT PRODUCTION OF SIRNAS IN SACCHAROMYCES BOULARDII AND PACKAGING IN EXTRACELLULAR VESICLES (EVs) FOR TARGETED GENE SILENCING

#686
20250051771
2025-02-13

MULTIVALENT CARGO-CARRYING COMPLEXES AND USES THEREOF

#687
20250051767
2025-02-13

iRNA Compositions and Methods for Silencing MYLIP

#688
20250051765
2025-02-13

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#689
20250049854
2025-02-13

CELLS COMPRISING A SUPPRESSOR OF GENE EXPRESSION AND/OR A SYNTHETICPATHWAY ACTIVATOR AND/OR AN INDUCIBLE PAYLOAD

#690
20250043291
2025-02-06

TRANSMISSIBLE ELEMENTS COMPRISING PATHWAY MODIFICATION SYSTEMS AND EXOGENOUS NUCLEIC ACIDS FOR THE PRODUCTION OF MOLECULES OF INTEREST

#691
20250043289
2025-02-06

3-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#692
20250043288
2025-02-06

PRODUCTS AND COMPOSITIONS

#693
20250043286
2025-02-06

METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE

#694
20250043282
2025-02-06

ATTENUATED ORTHOMYXOVIRUS-BASED VECTOR PLATFORM

#695
20250043281
2025-02-06

TREATMENT OF FGG RELATED DISEASES AND DISORDERS

#696
20250043279
2025-02-06

SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#697
20250041483
2025-02-06

GENETICALLY MODIFIED BIOPROSTHETIC HEART VALVE AND PRODUCTION METHOD THEREOF

#698
20250041423
2025-02-06

EXTRACTION OF PLANT SOURCE "MEDICINAL SOUP" AND MANUAL PREPARATION OF "HERBAL MEDICINE" AND RELATED PRODUCTS

#699
20250034578
2025-01-30

Subcutaneous Delivery of RNAi Agents for Inhibiting Expression of Receptor for Advanced Glycation End-products

#700
20250034577
2025-01-30

RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Compositions Thereof, and Methods of Use

#701
20250034576
2025-01-30

Double Stranded Oligonucleotide For Modulating JAK1 Expression

#702
20250034575
2025-01-30

OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS

#703
20250034573
2025-01-30

CIRCULAR RNA DERIVED FROM RNA VIRUSES AND RELATED COMPOSITIONS AND METHODS

#704
20250034572
2025-01-30

MODIFIED DOUBLE-STRANDED RNA AGENTS

#705
20250034571
2025-01-30

NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY

#706
20250034570
2025-01-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#707
20250034567
2025-01-30

CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#708
20250034566
2025-01-30

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#709
20250034565
2025-01-30

GLYCAN CONJUGATE COMPOSITIONS AND METHODS

#710
20250034561
2025-01-30

Novel Compositions for Conjugating Oligonucleotides and Carbohydrates

#711
20250032622
2025-01-30

COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES

#712
20250027111
2025-01-23

TEMPERATURE-BASED TRANSIENT DELIVERY OF NUCLEIC ACIDS AND PROTEINS TO CELLS AND TISSUES

#713
20250027105
2025-01-23

COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY

#714
20250027100
2025-01-23

USE OF MfERF026 GENE REGULATION IN GROWTH, DEVELOPMENT, AND STRESS TOLERANCE OF MEDICAGO SATIVA

#715
20250027091
2025-01-23

LIPID-PEGYLATED COMPOUNDS, PREPARATIONS AND USES THEREOF

#716
20250027086
2025-01-23

COMPOSITIONS AND METHODS FOR TREATMENT OF CANCERS USING MODIFIED siRNA-GEM AGENTS

#717
20250027085
2025-01-23

COMPOSITIONS AND METHODS FOR TREATING ALZHEIMER'S DISEASE UTILIZING A TRANSCRIPTIONAL MASTER REGULATOR OF THE RETROMER COMPLEX

#718
20250027082
2025-01-23

STAGGERED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS

#719
20250027054
2025-01-23

Compositions And Methods For Differentiation Of Human Pluripotent Stem Cells Into Desired Cell Types

#720
20250025570
2025-01-23

MUSCLE TARGETING COMPLEXES FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#721
20250025488
2025-01-23

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF TMPRSS6 AND IRON CHELATORS

#722
20250025478
2025-01-23

METHODS OF TARGETING RNF213 SIGNALING PATHWAY FOR TREATING DISEASES

#723
20250019763
2025-01-16

HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND MATURATION OF HUMAN DENDRITIC CELLS

#724
20250019709
2025-01-16

NOVEL OXO-RNA COMPOSITIONS AND THE RELATED APPLICATIONS THEREOF

#725
20250019708
2025-01-16

METHODS FOR THE TREATMENT OF HRD CANCER AND BRCA-ASSOCIATED CANCER

#726
20250019705
2025-01-16

PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING TARGET CANCER INCLUDING BRCA-SPECIFIC siRNA AS ACTIVE INGREDIENT

#727
20250019699
2025-01-16

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE

#728
20250019698
2025-01-16

IRNA COMPOSITIONS AND METHODS FOR SILENCING COMPLEMENT COMPONENT 3 (C3)

#729
20250019694
2025-01-16

TARGETING LIGAND AND USE THEREOF

#730
20250019668
2025-01-16

ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV)

#731
20250018045
2025-01-16

LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY

#732
20250018030
2025-01-16

PHARMACEUTICAL COMPOSITION FOR PROMOTING CANCER IMMUNOTHERAPY AND METHOD FOR PROMOTING CANCER IMMUNOTHERAPY

#733
20250011815
2025-01-09

AGENTS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS

#734
20250011802
2025-01-09

Methods for the Modification of Cells, Modified Cells and Uses Thereof

#735
20250011792
2025-01-09

IRAP INHIBITORS FOR USE IN THE TREATMENT OF INFLAMMATORY DISEASES

#736
20250011789
2025-01-09

Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof

#737
20250011788
2025-01-09

NUCLEIC ACID INTERFERENCE PHARMACEUTICAL COMPOSITION, AND DRUG FOR TREATING COLORECTAL CANCER, GASTRIC CANCER, AND PROSTATE CANCER

#738
20250011779
2025-01-09

COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS

#739
20250011778
2025-01-09

APP iRNA Compositions and Methods of Use Thereof for Treating or Preventing Diseases Characterized by Enlarged Endosomes

#740
20250011776
2025-01-09

HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#741
20250011751
2025-01-09

PROBES FOR DEPLETING ABUNDANT SMALL NONCODING RNA

#742
20250011404
2025-01-09

TARGETING APOE ENHANCES T-CELL KILLING IN CANCER IMMUNOTHERAPY

#743
20250009903
2025-01-09

PEPTIDE-BINDING HYBRID LIPOSOME EXOSOME, PEPTIDE-BINDING EXOSOME, COMPOSITION CONTAINING SAME, AND METHOD OF FORMING SAME

#744
20250009836
2025-01-09

COMPOSITIONS AND METHODS OF ALLEVIATING RESISTANCE TO CHEMOTHERAPY

#745
20250009740
2025-01-09

METHODS AND COMPOSITIONS FOR TARGETING ALTERNATIVE METABOLISM ALONG WITH FLT3 INHIBITOR-MEDIATED ANTILEUKEMIC ACTIONS

#746
20250009675
2025-01-09

PHOTO-CROSSLINKED BIOREDUCIBLE POLYMERIC NANOPARTICLES FOR ENHANCED RNA DELIVERY

#747
20250003969
2025-01-02

METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESISTANT INFLAMMATORY DISEASES

#748
20250002920
2025-01-02

GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS

#749
20250002918
2025-01-02

COMPOSITIONS AND METHODS FOR TREATMENT OF MIC60 DEPLETED CANCERS AND METASTASIS

#750
20250002916
2025-01-02

COMPOSITION FOR DIAGNOSIS, PREVENTION, OR TREATMENT OF VASCULAR SMOOTH MUSCLE CELL PROLIFERATIVE DISEASE, USING MIRNA INHIBITOR

#751
20250002913
2025-01-02

NUCLEIC ACIDS CONTAINING ABASIC NUCLEOSIDES

#752
20250002910
2025-01-02

TREATMENT OF COMPLEMENT-MEDIATED DISORDERS

#753
20250002908
2025-01-02

COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT COMPONENT 3 EXPRESSION

#754
20250002857
2025-01-02

Composition for inducing direct reprogramming comprising self-assembled RNA construct

#755
20250002488
2025-01-02

Glioblastoma Multiforme Treatments

#756
20250001005
2025-01-02

BLOCK COPOLYMERS AND USES THEREOF

#757
20250001003
2025-01-02

Lipid nanoparticle compositions and uses thereof

#758
20240426844
2024-12-26

POLY-GA PROTEINS IN ALZHEIMER’S DISEASE

#759
20240425864
2024-12-26

ANTISENSE OLIGONUCLEOTIDES HAVING ONE OR MORE ABASIC UNITS

#760
20240425863
2024-12-26

USE OF PI3KC2B INHIBITORS FOR THE PRESERVATION OF VASCULAR ENDOTHELIAL CELL BARRIER INTEGRITY

#761
20240425862
2024-12-26

SIRNA STRUCTURES FOR HIGH ACTIVITY AND REDUCED OFF TARGET

#762
20240425860
2024-12-26

OLIGONUCLEOTIDES FOR SARS-CoV-2 MODULATION

#763
20240425859
2024-12-26

PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV

#764
20240425857
2024-12-26

Means and Methods for Chronic Wound Healing

#765
20240425856
2024-12-26

Compositions and Methods for Treating Cag Repeat Diseases

#766
20240425854
2024-12-26

KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#767
20240425853
2024-12-26

MODIFIED SMALL INTERFERING RNA MOLECULES WITH REDUCED OFF-TARGET EFFECTS

#768
20240424135
2024-12-26

Compositions For and Methods of Improving Viral Vectors

#769
20240424134
2024-12-26

PEPTIDE HAVING INDEPENDENTLY STABILIZED HYDROPHOBIC ALPHA HELIX, PEPTIDE COMPLEX COMPRISING SAME AND USES THEREOF

#770
20240424131
2024-12-26

TARGETING NANOPARTICLES FOR THERAPY

#771
20240424105
2024-12-26

NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS

#772
20240423953
2024-12-26

METHODS AND COMPOSITIONS FOR TARGETING SV2 PROTEINS FOR IMMUNE REGULATION

#773
20240417756
2024-12-19

Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription

#774
20240417735
2024-12-19

ORAL CODELIVERY OF 5-FLUOREURACIL AND Bcl2 siRNA TREATING STOMACH CANCER

#775
20240417724
2024-12-19

AN ANTI-INFLAMMATORY COMPOSITION AND A METHOD OF OBTAINING THE SAME

#776
20240417723
2024-12-19

OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION

#777
20240417681
2024-12-19

METHODS AND COMPOSITIONS FOR PROMOTING SURVIVAL & PROLIFERATION OF ENDOTHELIAL CELLS & STIMULATING ANGIOGENESIS

#778
20240415953
2024-12-19

ORAL THERAPEUTIC VACCINE COMPOSITIONS, METHODS AND TREATMENT OF COVID

#779
20240415868
2024-12-19

COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE

#780
20240415852
2024-12-19

ORAL CODELIVERY OF NAVITOCLAX AND Bcl2 siRNA TREATING GASTIC CANCER

#781
20240409945
2024-12-12

RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S SYNDROME

#782
20240409944
2024-12-12

COMPOSITIONS AND METHODS FOR THE INHIBITION OF TUMOR METASTASIS AND HORIZONTAL GENE TRANSFER

#783
20240409943
2024-12-12

iRNA Compositions and Methods for Targeting ANGPTL7

#784
20240409942
2024-12-12

MODIFIED DOUBLE-STRANDED RNA AGENTS

#785
20240409938
2024-12-12

LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF CENTRAL NERVOUS SYSTEM DISEASES

#786
20240409937
2024-12-12

RNAi TARGETING HNRNPH2 MISSENSE MUTATIONS FOR TREATMENT OF BAIN SYNDROME

#787
20240409936
2024-12-12

RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSOCIATED NEUROLOGICAL DISORDER

#788
20240409935
2024-12-12

Atg8ylation coordinates stress granule formation and mTOR inactivation in response to lysosomal damage

#789
20240409934
2024-12-12

FOXO1-TARGETED THERAPY FOR THE TREATMENT OF CANCER

#790
20240409933
2024-12-12

CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TREATING NEUROLOGICAL DISEASES

#791
20240409565
2024-12-12

POLYCATIONIC METHYL PHOSPHOLIPIDS FOR IMPROVED DELIVERY OF NUCLEIC ACIDS TO EUKARYOTIC CELLS

#792
20240408227
2024-12-12

Muscle targeting complexes and uses thereof for treating dystrophinopathies

#793
20240408033
2024-12-12

CELL-DERIVED NANOVESICLES FOR IN VIVO TRANSPORT AND DELIVERY OF THERAPEUTIC MATERIALS

#794
20240401061
2024-12-05

COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION

#795
20240401060
2024-12-05

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#796
20240401058
2024-12-05

METHOD OF REGULATING PULMONARY ARTERY VASCULAR REMODELING

#797
20240401057
2024-12-05

ADAMTS14 INHIBITION

#798
20240401056
2024-12-05

FACTOR XII (F12) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#799
20240401055
2024-12-05

INHIBITION OF NEUROFIBRILLARY TANGLES USING OLIGONUCLEOTIDES AGAINST CIRCULAR RNAS FROM THE MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) LOCUS

#800
20240401053
2024-12-05

Compositions and methods for inhibiting LPA expression

#801
20240401045
2024-12-05

ANGIOTENSINOGEN-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF

#802
20240401042
2024-12-05

TUMOR DELIVERY OF DENDRITIC OLIGONUCLEOTIDES

#803
20240401040
2024-12-05

IN VIVO DELIVERY OF OLIGONUCLEOTIDES

#804
20240401039
2024-12-05

Compounds and Methods for Reducing ATXN2 Expression

#805
20240401037
2024-12-05

AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#806
20240401012
2024-12-05

SGF29 AS A TARGET FOR HOX/MYC DRIVEN CANCERS

#807
20240398968
2024-12-05

Muscle targeting complexes and uses thereof for treating dystrophinopathies

#808
20240398804
2024-12-05

METHODS OF TREATING CANCER HAVING AN ACTIVE WNT/BETA-CATENIN PATHWAY

#809
20240398799
2024-12-05

COMPOSITIONS AND METHODS FOR GENERATING SYNTHETIC LETHALITY IN TUMORS

#810
20240398720
2024-12-05

CATIONIC POLYMERS

#811
20240392320
2024-11-28

METHODS FOR ALTERING GENE EXPRESSION FOR GENETIC DISORDERS

#812
20240392299
2024-11-28

TREATMENT OF MST1R RELATED DISEASES AND DISORDERS

#813
20240392296
2024-11-28

Treatment of MST1 related diseases and disorders

#814
20240392295
2024-11-28

TREATMENT OF MST1 RELATED DISEASES AND DISORDERS

#815
20240392292
2024-11-28

RNAi Agents for Inhibiting Expression of Coronavirus (CoV) Viral Genomes, Compositions Thereof, and Methods of Use

#816
20240392289
2024-11-28

LIGAND CONJUGATES FOR DELIVERY OF THERAPEUTICALLY ACTIVE AGENTS

#817
20240392041
2024-11-28

Site-Specific Crosslinking of Antibodies

#818
20240391985
2024-11-28

NKD2 AS TARGET FOR TREATING RENAL FIBROSIS

#819
20240391870
2024-11-28

IONIZABLE CATIONIC LIPIDS FOR RNA DELIVERY

#820
20240390494
2024-11-28

Gene-regulating compositions and methods for improved immunotherapy

#821
20240384304
2024-11-21

INHIBITOR OLIGONUCLEOTIDES AND METHODS OF USE THEREOF

#822
20240384274
2024-11-21

COMPOSITIONS FOR AND METHODS OF TREATING AND/OR PREVENTING GLUTARIC ACIDURIA TYPE-1

#823
20240384273
2024-11-21

HSD17B13-RELATED DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO

#824
20240384271
2024-11-21

TARGETED GENE THERAPY FOR DM-1 MYOTONIC DYSTROPHY

#825
20240384234
2024-11-21

Method For Promoting Differentiation Of Pluripotent Stem Cells By Reducing Undifferentiated State Thereof

#826
20240382609
2024-11-21

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#827
20240382605
2024-11-21

CONJUGATED OLIGONUCLEOTIDES AND USES THEREOF

#828
20240382513
2024-11-21

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR MODULATION OF GENES ASSOCIATED WITH MUSCLE HEALTH

#829
20240382425
2024-11-21

RNA binding and stabilising cationic liposome, its application and method of loading the liposome with emetine

#830
20240382424
2024-11-21

LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF

#831
20240381876
2024-11-21

PLANT VECTORS, COMPOSITIONS AND USES RELATING THERETO

#832
20240376477
2024-11-14

COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#833
20240376476
2024-11-14

NUCLEIC ACID TARGETING PROPROTEIN CONVERTASE SUBTILISIN/KEXIN 9 AND USES THEREOF

#834
20240376475
2024-11-14

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF ANGIOPOIETIN-LIKE 3 (ANGPTL3) PROTEIN

#835
20240376471
2024-11-14

Treatment of Liver Diseases With Cell Death Inducing DFFA Like Effector B (CIDEB) Inhibitors

#836
20240376440
2024-11-14

ENGINEERED PRODUCER CELL LINES AND METHODS OF MAKING AND USING THE SAME

#837
20240374623
2024-11-14

TKTL1 INHIBITORS FOR ANTIVIRAL THERAPY

#838
20240368657
2024-11-07

INCLUSION BODY MEDIATED METHOD FOR DOUBLE-STRANDED RNA PRODUCING

#839
20240368604
2024-11-07

IL-34 ANTISENSE AGENTS AND METHODS OF USING SAME

#840
20240368601
2024-11-07

NCOVSIRNA DRUG FOR TARGETED DELIVERY SHRNA by RBD, SYNTHESIS METHOD, AND APPLICATION THEREOF

#841
20240368600
2024-11-07

NOVEL COMPOUND AND APPLICATION THEREOF

#842
20240368599
2024-11-07

PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING CANCER, CONTAINING CD300C EXPRESSION INHIBITOR OR ACTIVITY INHIBITOR

#843
20240368594
2024-11-07

HUNTINGTIN (HTT) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#844
20240368271
2024-11-07

Targeting GPR65 for the Treatment of Cancer in Overweight and Obese Individuals

#845
20240366760
2024-11-07

ACTIVATION OF SURVIVIN-SPECIFIC IMMUNE RESPONSES USING DENDRITIC CELL DERIVED EXOSOMES

#846
20240366632
2024-11-07

METHODS FOR THE TREATMENT OF OCULAR ROSACEA

#847
20240366604
2024-11-07

SELECTIVE INHIBITORS OF ROCK2 FOR THE TREATMENT OF MUSCULAR DYSTROPHY

#848
20240360474
2024-10-31

SELF-INACTIVATING VECTORS FOR GENE EDITING

#849
20240360456
2024-10-31

SYNTHETIC RNAS AND USES THEREOF

#850
20240360454
2024-10-31

RENAL INJURY BIOMARKERS AS BIOMARKERS FOR ACUTE HEPATIC PORPHYRIA (AHP)

#851
20240360448
2024-10-31

LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF

#852
20240360445
2024-10-31

CANCER TREATMENT USING siRNA TO MODULATE EXPRESSION OF PRDM2/RIZ PROTEIN

#853
20240360444
2024-10-31

DENDRITIC CONJUGATES FOR THE BRAIN DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES

#854
20240360211
2024-10-31

TREATMENT OF FIBROSIS

#855
20240358855
2024-10-31

MULTIGENE CONSTRUCTS FOR TREATMENT OF AGE-RELATED MACULAR DEGENERATION AND OTHER COMPLEMENT DYSREGULATION-RELATED CONDITIONS

#856
20240358738
2024-10-31

EXTRAHEPATIC DELIVERY

#857
20240358721
2024-10-31

GASDERMIN-D INHIBITORS AND USES THEREOF FOR TREATING PULMONARY VASO-OCCLUSION

#858
20240358007
2024-10-31

High Efficiency Beef Cattle Having Modified ACTN3 Genes

#859
20240352468
2024-10-24

HAIRPIN NUCLEIC ACID COMPOSITION

#860
20240352464
2024-10-24

Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof

#861
20240352460
2024-10-24

SNRNA TARGETING USH2A PRE-MRNA AND APPLICATION THEREOF

#862
20240352459
2024-10-24

COMPOSITIONS AND METHODS FOR SIRNA TREATMENT OF MUSCULAR DYSTROPHY

#863
20240352458
2024-10-24

DOUBLE STRANDED NUCLEIC ACID COMPOUNDS INHIBITING ZPI

#864
20240352457
2024-10-24

CONTROL OF INSECT INFESTATION

#865
20240352414
2024-10-24

THREE-DIMENSIONAL DIRECT NEURONAL REPROGRAMMING TO MODEL ALZHEIMER'S DISEASE IN HUMAN NEURONS

#866
20240352120
2024-10-24

COSTIMULATORY B7-H1 IN RENAL CELL CARCINOMA PATIENTS: INDICATOR OF TUMOR AGGRESSIVENESS AND POTENTIAL THERAPEUTIC TARGET

#867
20240352106
2024-10-24

PHARMACEUTICAL COMPOSITIONS TARGETING IMMUNE-MEDIATED PROCESSES IN NEURODEGENERATIVE DISEASE

#868
20240350669
2024-10-24

INHIBITION OF KYNURENINE SYNTHESIS AND/OR SIGNALING TO TREAT LEUKEMIA AND MYELODYSPLASIA

#869
20240350581
2024-10-24

METHODS FOR TREATMENT OF NEURON DEGENERATION

#870
20240350553
2024-10-24

METHODS FOR MODULATING THE REGENERATIVE PHENOTYPE IN MAMMALIAN CELLS

#871
20240350526
2024-10-24

DENDRITIC CONJUGATES FOR THE SKIN DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES

#872
20240344073
2024-10-17

PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#873
20240344072
2024-10-17

TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS

#874
20240344071
2024-10-17

Products and Methods for Treatment of Amyotrophic Lateral Sclerosis

#875
20240344070
2024-10-17

METHODS AND COMPOSITIONS FOR TREATING SUBJECTS HAVING OR AT RISK OF DEVELOPING A NON-PRIMARY HYPEROXALURIA DISEASE OR DISORDER

#876
20240344068
2024-10-17

DUAL FUNCTION HYBRID NANOPARTICLES AND METHODS OF USING THE SAME TO TREAT DISEASES AND DISORDERS

#877
20240344063
2024-10-17

COMPOSITIONS AND METHODS FOR INHIBITING LPA EXPRESSION

#878
20240343828
2024-10-17

SPINK1 AS A TARGET FOR THERAPEUTIC INTERVENTION IN LUNG DISEASES

#879
20240343787
2024-10-17

METHODS FOR TREATING SICKLE CELL DISEASE OR BETA THALASSEMIA USING COMPLEMENT ALTERNATIVE PATHWAY INHIBITORS

#880
20240342312
2024-10-17

A SHORTENED P63-PROTEIN DOMAIN TO ENHANCE HUMAN CARDIAC REPROGRAMMING

#881
20240342179
2024-10-17

TREATMENT OF CANCERS OR NEOPLASMS BY INHIBITING KIF15

#882
20240342088
2024-10-17

CATIONIC LIPID, LIPOSOME CONTAINING CATIONIC LIPID, AND NUCLEIC-ACID PHARMACEUTICAL COMPOSITION CONTAINING LIPOSOME AND FORMULATION AND APPLICATION THEREOF

#883
20240336922
2024-10-10

INHIBITORS OF EXPRESSION AND/OR FUNCTION

#884
20240336921
2024-10-10

USE OF OLIGONUCLEOTIDES FOR INDIVIDUALS WITH RENAL IMPAIRMENT

#885
20240336918
2024-10-10

METHODS OF CONTROLLING RNA BINDING PROTEIN ACTIVITY

#886
20240336917
2024-10-10

COMPOSITIONS AND METHODS FOR INHIBITING THE EXPRESSION OF TMIGD2

#887
20240336915
2024-10-10

COMPOUNDS AND METHODS FOR REDUCING DUX4 EXPRESSION

#888
20240336914
2024-10-10

2'-MODIFIED NUCLEOSIDE BASED OLIGONUCLEOTIDE PRODRUGS

#889
20240335505
2024-10-10

PRODUCTS AND METHODS FOR PROMOTING MYOGENESIS

#890
20240335465
2024-10-10

A NON-CANONICAL SIGNALING ACTIVITY OF CGAMP TRIGGERS DNA DAMAGE RESPONSE SIGNALING

#891
20240327845
2024-10-03

ANTISENSE OLIGONUCLEOTIDES TARGETING UNC13A

#892
20240327843
2024-10-03

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL

#893
20240327842
2024-10-03

GALNAC-MONOMERS AND GALNAC-NUCLEIC ACID CONJUGATES

#894
20240327841
2024-10-03

COMPOSITIONS COMPRISING DOPED SILICON PARTICLES, AND RELATED METHODS

#895
20240327839
2024-10-03

NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF

#896
20240327838
2024-10-03

MODULATORS OF ENaC EXPRESSION

#897
20240327836
2024-10-03

MODIFIED OLIGONUCLEOTIDES TARGETING SNPs

#898
20240327835
2024-10-03

METHODS FOR REACTIVATING GENES ON THE INACTIVE X CHROMOSOME

#899
20240327834
2024-10-03

LIPID FORMULATED COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF SERUM AMYLOID A GENE

#900
20240327832
2024-10-03

NUCLEIC ACID CONSTRUCT ENABLING EXPRESSION AND INHIBITION OF GENE SIMULTANEOUSLY