ClassID:

109145

C12N2310/14 - page 6 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.

Recent Application in this class:
#1501
20230233535
2023-07-27

Selective inhibition of T follicular helper cells for treatment of autoimmune disorders

#1502
20230227830
2023-07-20

METHODS AND COMPOSITIONS OF RNA NANOSTRUCTURES FOR REPLICATION AND SUB-GENOMIC EXPRESSION BY RNA-DIRECTED RNA POLYMERASE

#1503
20230227583
2023-07-20

COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS

#1504
20230226193
2023-07-20

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS

#1505
20230226180
2023-07-20

METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS

#1506
20230226148
2023-07-20

METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS

#1507
20230220398
2023-07-13

COMPOSITIONS AND METHODS FOR INHIBITING NUCLEAR RECEPTOR SUBFAMILY 1 GROUP H MEMBER 3 (NR1H3) EXPRESSION

#1508
20230220396
2023-07-13

Transmembrane protease, serine 6 (TMPRSS6) iRNA compositions and methods of use thereof

#1509
20230220393
2023-07-13

METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT

#1510
20230220391
2023-07-13

CILP-1 Inhibitors for Use in the Treatment of Dilated Cardiomyopathies

#1511
20230220388
2023-07-13

MULTIMERIC OLIGONUCLEOTIDES WITH DIVIDED STRANDS

#1512
20230220387
2023-07-13

D-SERINE TRANSPORT MODIFIER AND SCREENING METHOD THEREOF, AND SCREENING METHOD OF D-SERINE TRANSPORTER PROTEIN

#1513
20230220384
2023-07-13

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

#1514
20230220380
2023-07-13

GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY

#1515
20230212614
2023-07-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA DIRECTED MODULATION OF TRANSCRIPTION

#1516
20230212585
2023-07-06

Cellular Ablation of HLA-Class I MHC

#1517
20230212584
2023-07-06

MEDICAMENT USED FOR TREATING CHOLANGIOCARCINOMA WITH KRAS MUTATIONS

#1518
20230212581
2023-07-06

COMPOSITIONS AND METHODS OF INDUCING RNAI OR TYPE I IFN COMPETENT CELLS AND USES THEREOF

#1519
20230212578
2023-07-06

COMPOSITIONS AND METHODS FOR TREATING HYPERTRIGLYCERIDEMIA

#1520
20230212576
2023-07-06

MAPT RNA INTERFERENCE AGENTS

#1521
20230210971
2023-07-06

EDIBLE PLANT EXOSOME-LIKE NANOVECTORS FOR VACCINATION

#1522
20230210887
2023-07-06

NUCLEIC ACID MOLECULES FOR REDUCTION OF PAPD5 OR PAPD7 MRNA FOR TREATING HEPATITIS B INFECTION

#1523
20230210106
2023-07-06

RNAi FOR CONTROL OF PHLOEM SAP-FEEDING INSECTS IN CROP PLANTS

#1524
20230203500
2023-06-29

GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS

#1525
20230203499
2023-06-29

SYSTEMS AND METHODS FOR TREATING LEVODOPA DYSKINESIA, ENHANCING MOTOR BENEFIT, AND DELAYING DISEASE PROGRESSION

#1526
20230203497
2023-06-29

DYNAMIN 2 INHIBITOR FOR THE TREATMENT OF CENTRONUCLEAR MYOPATHIES

#1527
20230203495
2023-06-29

FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE SKIN GRAFT HEALING

#1528
20230203494
2023-06-29

AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME

#1529
20230203493
2023-06-29

Biomarkers Related to Oral Squamous Cell Carcinoma and Methods of Diagnosis and Treatment Thereof

#1530
20230203491
2023-06-29

DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR TREATING COVID-19 CONTAINING SAME

#1531
20230203490
2023-06-29

UTILIZING RNA INTERFERENCE AGAINST SARS-COV-2

#1532
20230203489
2023-06-29

COMPOSITIONS AND METHODS FOR CONTROLLING LEPTINOTARSA

#1533
20230203487
2023-06-29

EXOSOME-DERIVED PIWI-INTERACTING RNA AND METHODS OF USE THEREOF

#1534
20230203486
2023-06-29

MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1535
20230203484
2023-06-29

DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO

#1536
20230203180
2023-06-29

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR MODULATION OF GENES ASSOCIATED WITH MUSCLE HEALTH

#1537
20230203137
2023-06-29

PREPARATION METHOD OF ARTIFICIAL ANTIBODY

#1538
20230203085
2023-06-29

MULTI-CONJUGATES COMPRISING MULTIPLE LIGANDS

#1539
20230203078
2023-06-29

SYNTHESIS OF 3'N NUCLEOSIDES THROUGH OXIME INTERMEDIATES AND RELATED COMPOUNDS

#1540
20230201363
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#1541
20230201362
2023-06-29

Compositions and methods of treating muscle atrophy and myotonic dystrophy

#1542
20230201358
2023-06-29

LINKER COMPOUNDS

#1543
20230201243
2023-06-29

MODULATORS OF FOXP3 EXPRESSION

#1544
20230193284
2023-06-22

TRANSMEMBRANE SERINE PROTEASE 2 (TMPRSS2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1545
20230193283
2023-06-22

COMPOSITION FOR PREVENTING OR TREATING DISEASE CAUSED BY MUSCLE LOSS, COMPRISING AGENT INHIBITING PHF20

#1546
20230193281
2023-06-22

OLIGONUCLEOTIDES FOR SOD1 MODULATION

#1547
20230193278
2023-06-22

MULTI-TARGETED siRNA FOR TREATING CANCERS

#1548
20230193277
2023-06-22

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#1549
20230193276
2023-06-22

Composition of drug targets and method of using thereof

#1550
20230193268
2023-06-22

APOLIPOPROTEIN E (APOE) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1551
20230193267
2023-06-22

CARDIAC CELL PROLIFERATION BY ADMINISTERING INHIBITORS OF SAV1, NF2, MOB1 AND/OR MUTANT SRF

#1552
20230193259
2023-06-22

COMPOUNDS AND METHODS FOR THE TREATMENT OF CANCER

#1553
20230192879
2023-06-22

METHODS FOR THE DIAGNOSIS AND TREATMENT OF CYTOKINE RELEASE SYNDROME

#1554
20230192874
2023-06-22

Human antibodies to the human glucagon receptor (HGCGR) and methods of use thereof to lower blood glucose or ketone levels

#1555
20230192783
2023-06-22

RECOMBINANT POLYPEPTIDES FOR MEMBRANE FUSION AND USES THEREOF

#1556
20230190963
2023-06-22

Treating metastatic cancer and model systems for metastatic disease

#1557
20230190962
2023-06-22

METHODS FOR TREATING GAIN-OF-FUNCTION DISORDERS COMBINING GENE EDITING AND GENE THERAPY

#1558
20230190753
2023-06-22

COMPOSITIONS AND METHODS FOR THE TREATMENT OF A BETA-CATENIN-ASSOCIATED DISEASE OR DISORDER

#1559
20230189819
2023-06-22

COMPOSITIONS AND METHODS FOR FUNGAL INHIBITION USING MINICELL-BASED RNAi

#1560
20230183746
2023-06-15

COMPOSITIONS FOR TRANSFER OF CARGO TO CELLS

#1561
20230183707
2023-06-15

COMPOSITIONS AND METHODS FOR INHIBITING MARC1 GENE EXPRESSION

#1562
20230183705
2023-06-15

PRODUCTS FOR SUPPRESSING OR REDUCING THE EXPRESSION OR ACTIVITY OF A SNORNA AND USES THEREOF IN THE TREATMENT OF CANCER

#1563
20230183701
2023-06-15

Modified double-stranded RNA agents

#1564
20230183695
2023-06-15

COMPOSITIONS AND METHODS FOR THE DELIVERY OF AGENTS TO BIOLOGICAL TARGETS

#1565
20230181528
2023-06-15

COMPOSITIONS AND METHODS FOR TREATING NEOPLASIA

#1566
20230181467
2023-06-15

Hybridosomes, compositions comprising the same, processes for their production and uses thereof

#1567
20230175009
2023-06-08

IMMUNOLOGICALLY COMPATIBLE AND REVERSIBLE UNIVERSAL PLURIPOTENT STEM CELL AND APPLICATION THEREOF

#1568
20230174988
2023-06-08

METHODS FOR INDUCING BILE ACID SULFOTRANSFERASE SULT2A FOR TREATING METABOLIC DISORDERS

#1569
20230174986
2023-06-08

Medication and diagnostic kit for inhibiting metastasis and invasion of breast cancer, shRNA molecule for silencing expression of human LINC01614 and application thereof

#1570
20230174978
2023-06-08

METHODS AND COMPOSITIONS FOR MODULATING GENE EXPRESSION

#1571
20230173096
2023-06-08

TARGETED ANTIVIRAL DRUGS

#1572
20230167449
2023-06-01

DEPLETION OF EXT1 EXPRESSION AND/OR ACTIVITY IMPROVES CELLULAR PRODUCTION OF BIOLOGICAL ENTITIES

#1573
20230167446
2023-06-01

COMPOUNDS AND METHODS FOR REDUCING PSD3 EXPRESSION

#1574
20230167444
2023-06-01

COMPOSITIONS AND METHODS FOR INTRANASAL TREATMENT WITH DOUBLE STRANDED RNA

#1575
20230167440
2023-06-01

METHOD OF STIMULATING PROLIFERATION OF A CELL

#1576
20230159933
2023-05-25

COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION

#1577
20230159931
2023-05-25

TARGETING THE PALMOTYLATION/DEPALMOTYLATION CYCLE TO TREAT INFLAMMATORY DISEASES

#1578
20230159929
2023-05-25

MODIFIED SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF

#1579
20230159918
2023-05-25

USE OF LNCRNA XR_595534.2 IN PREPARATION OF MEDICINE FOR TREATMENT OR PREVENTION OF CHRONIC PAIN

#1580
20230159650
2023-05-25

Composition for preventing or treating diseases caused by overexpression of chemokine CXCL1, containing death receptor inhibitor as active ingredient

#1581
20230159625
2023-05-25

EXPRESSION OF FC-CONTAINING PROTEINS

#1582
20230158150
2023-05-25

COMPOUND COMPRISING A NUCLEIC ACID AND A HALF-LIFE EXTENSION MOTIF

#1583
20230158059
2023-05-25

Prekallikrein-modulating compositions and methods of use thereof

#1584
20230151370
2023-05-18

METHODS AND COMPOSITIONS FOR APTAMER-DRIVEN SURFACE FORMULATION OF SELF-FORMING POLYNUCLEOTIDE NANOPARTICLES

#1585
20230151369
2023-05-18

COMPOSITIONS AND METHODS FOR INHIBITING TDP-43 AND FUS AGGREGATION

#1586
20230151368
2023-05-18

EXTRACELLULAR VESICLE SECRETION REDUCING AGENT FOR REDUCING EXTRACELLULAR VESICLE SECRETION, AND USE OF THE SAME

#1587
20230151363
2023-05-18

MODIFIED SHORT-INTERFERING RNA COMPOSITIONS AND THEIR USE IN THE TREATMENT OF CANCER

#1588
20230151118
2023-05-18

ARTC1 LIGANDS FOR CANCER TREATMENT

#1589
20230151084
2023-05-18

COMPOSITIONS AND METHODS OF MODULATING B CELL RESPONSE

#1590
20230149507
2023-05-18

TREATMENT OF ALT CANCERS

#1591
20230149437
2023-05-18

METHODS FOR ENHANCING VASCULAR DENSITY

#1592
20230147979
2023-05-11

DESIGN METHOD FOR OPTIMIZED RIG-I LIGANDS

#1593
20230146956
2023-05-11

MULTIMERIC OLIGONUCLEOTIDES WITH DIVIDED STRANDS

#1594
20230144739
2023-05-11

TREATMENT OF COVID-19 WITH REVERSE MICELLE SYSTEM COMPRISING UNMODIFIED OLIGONUCLEOTIDES

#1595
20230144623
2023-05-11

SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY

#1596
20230141929
2023-05-11

METHOD FOR TREATING CARDIOVASCULAR DISEASE

#1597
20230141417
2023-05-11

METHODS AND COMPOSITIONS FOR INACTIVATING INTERLEUKIN-2-INDUCIBLE T-CELL KINASE (ITK)

#1598
20230139322
2023-05-04

SiRNA molecule inhibiting the expression of the PCSK9 gene and use thereof

#1599
20230139166
2023-05-04

RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use

#1600
20230138928
2023-05-04

1'-ALKYL MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE

#1601
20230138507
2023-05-04

ALPHA-2A ADRENERGIC RECEPTOR (ADRA2A) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1602
20230138103
2023-05-04

GENE SILENCING AGENTS FOR TARGETING CORONAVIRUS GENES AND USES THEREOF

#1603
20230136787
2023-05-04

COMPOSITIONS AND METHODS FOR SILENCING VEGF-A EXPRESSION

#1604
20230135763
2023-05-04

PRODUCTS AND COMPOSITIONS

#1605
20230133637
2023-05-04

ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1606
20230132756
2023-05-04

DOUBLE-STRANDED OLIGONUCLEOTIDE, COMPOSITION AND CONJUGATE COMPRISING DOUBLE-STRANDED OLIGONUCLEOTIDE, PREPARATION METHOD THEREOF AND USE THEREOF

#1607
20230132275
2023-04-27

USE OF CDON INHIBITORS FOR THE TREATMENT OF ENDOTHELIAL DYSFUNCTION

#1608
20230131243
2023-04-27

METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1

#1609
20230129386
2023-04-27

TREATMENT OF COVID-19 WITH REVERSE MICELLE SYSTEM COMPRISING UNMODIFIED OLIGONUCLEOTIDES

#1610
20230126881
2023-04-27

Fc FRAGMENT OF IgG RECEPTOR AND TRANSPORTER (FCGRT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1611
20230126233
2023-04-27

LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1612
20230125933
2023-04-27

MANNAN BINDING LECTIN SERINE PEPTIDASE 2 (MASP2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1613
20230125671
2023-04-27

RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use

#1614
20230124032
2023-04-20

Composition for preventing or treating keloids or hypertrophic scars

#1615
20230123981
2023-04-20

4'-O-METHYLENE PHOSPHONATE NUCLEIC ACIDS AND ANALOGUES THEREOF

#1616
20230123754
2023-04-20

RNA-DIRECTED DNA CLEAVAGE BY THE Cas9-crRNA COMPLEX

#1617
20230123513
2023-04-20

Deaminase-based RNA sensors

#1618
20230123192
2023-04-20

ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1619
20230123187
2023-04-20

METHODS AND COMPOSITIONS FOR TREATMENT OF ATHEROSCLEROSIS

#1620
20230122801
2023-04-20

USP10 TARGETED SELF-DELIVERABLE SIRNA COMPOSITIONS AND METHODS FOR PREVENTING OR INHIBITING FIBROSIS AND/OR SCARRING

#1621
20230122751
2023-04-20

USE OF COPS3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION

#1622
20230122244
2023-04-20

CHIRALLY-ENRICHED DOUBLE-STRANDED RNA AGENTS

#1623
20230121944
2023-04-20

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION

#1624
20230121917
2023-04-20

Immunomodulatory RNA

#1625
20230121720
2023-04-20

DIAGNOSTIC METHODS USING PCG-1A EXPRESSION

#1626
20230120244
2023-04-20

HYPERBRANCHED POLYMERS AND POLYPLEXES AND DNA OR RNA DELIVERY SYSTEMS INCLUDING THE SAME

#1627
20230120063
2023-04-20

USE OF SARAF INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION

#1628
20230119344
2023-04-20

RNAI INDUCED HUNTINGTIN GENE SUPPRESSION

#1629
20230118799
2023-04-20

Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy

#1630
20230118138
2023-04-20

USE OF SCAMP3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION

#1631
20230117883
2023-04-20

MUSCLE-TARGETING COMPLEXES AND USES THEREOF IN TREATING MUSCLE ATROPHY

#1632
20230116019
2023-04-13

NANOPARTICLES FOR EXPRESSION OF GENES OF INTEREST AND/OR REGULATION OF SIGNALING PATHWAYS

#1633
20230114649
2023-04-13

HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1634
20230113948
2023-04-13

SYNTHETIC PROCESSES AND INTERMEDIATES

#1635
20230113866
2023-04-13

Methods Of Treating Clonal Hematopoiesis Of Indeterminate Potential (CHIP) With Lymphocyte Antigen 75 (LY75), Cluster Of Differentiation 164 (CD164), Or Poly(ADP-Ribose) Polymerase 1 (PARP1) Inhibitors

#1636
20230111150
2023-04-13

METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF KRAS BY ASYMMETRIC DOUBLE-STRANDED RNA

#1637
20230110876
2023-04-13

MODIFIED DOUBLE-STRANDED RNA AGENTS

#1638
20230110295
2023-04-13

Targeted compositions

#1639
20230110095
2023-04-13

Compound and application thereof

#1640
20230109183
2023-04-06

TRIALKYL CATIONIC LIPIDS AND METHODS OF USE THEREOF

#1641
20230108340
2023-04-06

METHODS FOR REDUCING HTT EXPRESSION

#1642
20230107967
2023-04-06

COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-1 ANTITRYPSIN EXPRESSION

#1643
20230107757
2023-04-06

POLY(BETA-AMINO ESTER)-CO-POLYETHYLENE GLYCOL (PEG-PBAE-PEG) POLYMERS FOR GENE AND DRUG DELIVERY

#1644
20230107173
2023-04-06

Methods Of Treating Chronic Kidney Disease (CKD) With Inhibitors Of Protective Loss-Of-Function Genes

#1645
20230104125
2023-04-06

METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER

#1646
20230103549
2023-04-06

OVERLAPPING THERAPEUTIC STRATEGIES FOR CYSTINOSIS TREATMENT AND COSMETIC SKIN DARKENING

#1647
20230101828
2023-03-30

KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1648
20230101807
2023-03-30

Increasing gene expression

#1649
20230101227
2023-03-30

Compositions comprising reversibly modified oligonucleotides and uses thereof

#1650
20230099879
2023-03-30

Cancer treatment using siRNA to modulate expression of PRDM2/RIZ protein

#1651
20230099109
2023-03-30

Treatment Of Glaucoma With Rho Guanine Nucleotide Exchange Factor 12 (ARHGEF12) Inhibitors

#1652
20230099101
2023-03-30

SERINE PROTEASE INHIBITORS FOR SUPPRESSING OR PREVENTING ANAPHYLACTIC REACTION

#1653
20230098307
2023-03-30

VITAMIN B6-COUPLED POLYOL-BASED POLYDIXYLITOL GENE TRANSPORTER COMPRISING PEPTIDE BINDING SPECIFICALLY TO CANCER STEM CELL AND CANCER STEM CELL-TARGETED THERAPY TECHNIQUE

#1654
20230095566
2023-03-30

ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS

#1655
20230093948
2023-03-30

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1656
20230093888
2023-03-30

Compositions and methods for delivery of nucleic acids to cells

#1657
20230093238
2023-03-23

Methods of treating cancers having a BRCA1 and/or BRCA2 mutation(s)

#1658
20230092615
2023-03-23

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSING OF METHYLATION-CONTROLLED J-PROTEIN (MCJ)

#1659
20230089915
2023-03-23

PRODUCTS AND COMPOSITIONS

#1660
20230089478
2023-03-23

CHEMICALLY MODIFIED OLIGONUCLEOTIDES WITH IMPROVED SYSTEMIC DELIVERY

#1661
20230089224
2023-03-23

Targeted therapy composition and its use for suppressing breast cancer cell proliferation, migration or invasion

#1662
20230087487
2023-03-23

TOPICAL DELIVERY OF RNA INTERFERENCE AGENTS USING IONIC LIQUID

#1663
20230085308
2023-03-16

Compositions and methods for delivery of nucleic acids to cells

#1664
20230085277
2023-03-16

Adeno-associated virus for activating RNA-NEAT1 over-expression and applications thereof

#1665
20230082311
2023-03-16

DRUG FOR CURATIVE THERAPY OF INTRACTABLE HEREDITARY RENAL ALPORT SYNDROME

#1666
20230080252
2023-03-16

ANTICANCER ADJUVANT AND PHARMACEUTICAL COMPOSITION FOR TREATING ANTICANCER-AGENT-RESISTANT CANCER, AND KIT COMPRISING SAME

#1667
20230079757
2023-03-16

METHODS AND MATERIALS FOR TREATING CANCER

#1668
20230079754
2023-03-16

Methods and compositions for reducing pathogenic isoforms

#1669
20230079745
2023-03-16

COMPOSITIONS COMPRISING BACTERIALLY DERIVED MINICELLS AND METHODS OF USING THE SAME

#1670
20230078200
2023-03-16

RNAi CONSTRUCTS AND METHODS FOR INHIBITING LPA EXPRESSION

#1671
20230076063
2023-03-09

COMPOSITIONS AND METHODS FOR TREATING OR AMELIORATING A MYCOBACTERIUM TUBERCULOSIS INFECTION

#1672
20230075981
2023-03-09

Composition for preventing or treating cognitive dysfunction including inhibitor or MECP2 expression

#1673
20230075314
2023-03-09

VECTORIZED ANTIBODIES (vAb) AND USES THEREOF

#1674
20230074721
2023-03-09

Treatment Of Inflammatory Diseases With RAS Protein Activator Like 3 (RASAL3) Inhibitors

#1675
20230074280
2023-03-09

TREATMENT OF THYMIC STROMAL LYMPHOPOIETIN (TSLP) RELATED DISEASES BY INHIBITION OF LONG-FORM TSLP TRANSCRIPTS

#1676
20230073368
2023-03-09

THERAPY OF RAS-DEPENDENT CANCERS

#1677
20230070477
2023-03-09

REPROGRAMMING THE METABOLOME TO DELAY ONSET OR TREAT NEURODEGENERATION

#1678
20230070118
2023-03-09

Multi-conjugate of siRNA and preparing method thereof

#1679
20230069235
2023-03-02

METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF ALPHA-1 ANTITRYPSIN BY DOUBLE-STRANDED RNA

#1680
20230068339
2023-03-02

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1681
20230067484
2023-03-02

Methods and compositions for genomic integration

#1682
20230066830
2023-03-02

METHODS AND COMPOSITIONS FOR INDUCING APOPTOSIS IN CANCER STEM CELLS

#1683
20230066380
2023-03-02

ANTAGONISM AS A THERAPY FOR TDP-43 PROTEINOPATHIES

#1684
20230066056
2023-03-02

METHODS AND USES FOR PROPROTEIN CONVERTASE SUBTILISIN KEXIN 9 (PCSK9) INHIBITORS

#1685
20230065782
2023-03-02

TARGETED AND LOCALIZED IN VIVO DELIVERY OF OLIGONUCLEOTIDES

#1686
20230064031
2023-03-02

4′-phosphate analogs and oligonucleotides comprising the same

#1687
20230063922
2023-03-02

RIBONUCLEOPROTEINS FOR RNA THERAPEUTICS DELIVERY AND GENE SILENCING

#1688
20230062603
2023-03-02

FORMULATIONS FOR DELIVERY OF OLIGONUCLEOTIDES TO LUNG CELLS

#1689
20230059929
2023-02-23

Modulation Of Endoplasmic Reticulum Aminopeptidase 2 (ERAP2)-Mediated Immune Response

#1690
20230058834
2023-02-23

Methods and compositions for the specific inhibition of transthyretin (TTR) by double-stranded RNA

#1691
20230057430
2023-02-23

INHIBITION OF TAP63 REGULATED ONCOGENIC LONG NON-CODING RNAS (TROLLS) IN THE TREATMENT OF CANCER

#1692
20230056788
2023-02-23

METHODS AND COMPOSITIONS FOR THE INHIBITION OF HEPATITIS B AND HEPATITIS D VIRUS INFECTIONS

#1693
20230056569
2023-02-23

ATAXIN3 (ATXN3) RNAI AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#1694
20230056466
2023-02-23

NOVEL PRECURSOR MIRNA AND APPLICATION THEREOF IN TUMOR TREATMENT

#1695
20230055912
2023-02-23

Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors

#1696
20230055405
2023-02-23

COMPOUNDS AND METHODS FOR REDUCING APP EXPRESSION

#1697
20230054941
2023-02-23

INHIBITION OF DENND5B EXPRESSION FOR TREATING HEPATIC STEATOSIS

#1698
20230054672
2023-02-23

METHODS AND COMPOSITIONS FOR MODULATING GENE EXPRESSION

#1699
20230053332
2023-02-23

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

#1700
20230050684
2023-02-16

USE OF POTASSIUM CHANNEL INHIBITOR FOR TREATING DEPRESSION

#1701
20230049529
2023-02-16

MODIFIED DOUBLE STRANDED OLIGONUCLEOTIDE

#1702
20230048730
2023-02-16

PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF

#1703
20230048681
2023-02-16

COMPOSITIONS AND METHODS OF TREATMENT FOR LYTIC AND LYSOGENIC VIRUSES

#1704
20230047754
2023-02-16

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#1705
20230047473
2023-02-16

siRNA based on RNA sequence of SARS-CoV-2 and use thereof

#1706
20230047351
2023-02-16

System for the biocontrol of white spot syndrome virus (WSSV) in aquaculture

#1707
20230045629
2023-02-09

TREATMENT OF PROGRESSIVE SUPRANUCLEAR PALSY

#1708
20230045314
2023-02-09

Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy

#1709
20230043964
2023-02-09

METHODS AND COMPOSITIONS FOR TREATING ATHEROSCLEROSIS

#1710
20230042493
2023-02-09

CTGF GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE, AND A COMPOSITION FOR PREVENTING AND TREATING FIBROTIC DISEASES AND RESPIRATORY-RELATED DISEASES COMPRISING SAME

#1711
20230042451
2023-02-09

Compositions and methods for inhibiting mitochondria amidoxime reducing component 1 (MARC1) expression

#1712
20230042446
2023-02-09

ADOPTIVE CELL THERAPY WITH ZBTB20 SUPPRESSION

#1713
20230042198
2023-02-09

Methods and Compositions for Modulationg Heterochromatin Dysfunction, Genomic Instability, and Associate Conditions

#1714
20230042176
2023-02-09

METHOD FOR TREATING ANGELMAN SYNDROME AND RELATED DISORDERS

#1715
20230040920
2023-02-09

COMPOSITIONS AND METHODS FOR SILENCING DNAJB1-PRKACA FUSION GENE EXPRESSION

#1716
20230039520
2023-02-09

PERICYTE-SPARING THERAPY

#1717
20230039443
2023-02-09

PROCESS FOR BUILDING NANOPARTICLE-BASED DRUG CARRIERS VIA PROTEIN CORONA MODULATION

#1718
20230039169
2023-02-09

Modified EC7 Cells Having Low Toxicity to Viral Production Payloads

#1719
20230038503
2023-02-09

INHIBITORS OF KDM5A FOR USE IN TREATMENT OF IDIOPATHIC INFLAMMATORY MYOPATHIES

#1720
20230037582
2023-02-09

Treatment Of Psoriasis With Interferon Induced Helicase C Domain 1 (IFIH1) Inhibitors

#1721
20230036569
2023-02-02

ENGINEERED IMMUNE CELLS WITH REDUCED TOXICITY AND USES THEREOF

#1722
20230035774
2023-02-02

Compositions and methods for treating cancer

#1723
20230034732
2023-02-02

Targeting cell tropism receptors to inhibit cytomegalovirus infection

#1724
20230034093
2023-02-02

Treatment Of Cognitive Impairment With Alpha-N-Acetylgalactosaminide Alpha-2,6-Sialyltransferase 5 (ST6GALNAC5) Inhibitors

#1725
20230032060
2023-02-02

Compositions and methods for delivery of nucleic acids to cells

#1726
20230031669
2023-02-02

HSD17B13 VARIANTS AND USES THEREOF

#1727
20230031499
2023-02-02

TARGETING GLIOBLASTOMA STEM CELLS THROUGH THE TLX-TET3 AXIS

#1728
20230030119
2023-02-02

RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)

#1729
20230029377
2023-01-26

METHODS AND COMPOSITIONS TO PROMOTING RETINAL REGENERATION USING PROX1 MIGRATION INHIBITOR AS ACTIVE INGREDIENT

#1730
20230029227
2023-01-26

Tunable Reversir™ compounds

#1731
20230028937
2023-01-26

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

#1732
20230027604
2023-01-26

APOLIPOPROTEIN B ANTAGONIST

#1733
20230027007
2023-01-26

Treatment of Hypertension With Solute Carrier Family 9 Isoform A3 Regulatory Factor 2 (SLC9A3R2) Inhibitors

#1734
20230026968
2023-01-26

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#1735
20230026844
2023-01-26

Inhibitors of Cancer Biomarkers and Uses Thereof

#1736
20230026843
2023-01-26

Compositions and methods for organ specific delivery of nucleic acids

#1737
20230025910
2023-01-26

Compounds and methods for reducing IFNAR1 expression

#1738
20230024926
2023-01-26

Nucleic acids for inhibiting expression of C3 in a cell

#1739
20230024849
2023-01-26

NEUROFILAMENT LIGHT CHAIN (NFL) AS A BIOMARKER FOR TRANSTHYRETIN AMYLOIDOSIS POLYNEUROPATHY

#1740
20230022590
2023-01-26

NOVEL RNA THERAPEUTICS AND USES THEREOF

#1741
20230022185
2023-01-26

Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases

#1742
20230021840
2023-01-26

USE OF GP73 INHIBITOR IN PREPARATION OF MEDICINE FOR TREATING DIABETES

#1743
20230021584
2023-01-26

Methods Of Treating Decreased Bone Mineral Density With Kringle Containing Transmembrane Protein 1 (KREMEN1) Inhibitors

#1744
20230021431
2023-01-26

Oligonucleotides for SARS-CoV-2 modulation

#1745
20230020545
2023-01-19

Methods for reactivating genes on the inactive X chromosome

#1746
20230020192
2023-01-19

COMPOUNDS AND METHODS FOR MODULATING C90RF72

#1747
20230019513
2023-01-19

Nucleic acids for inhibiting expression of PROS1 in a cell

#1748
20230018989
2023-01-19

INHIBITING THE RNA METHYLTRANSFERASE METTL3 OR ITS INTERACTION WITH EIF3H TO SUPPRESS ONCOGENE TRANSLATION AND TUMORIGENESIS

#1749
20230017666
2023-01-19

AN UBIQUITIN LIGASE INHIBITOR FOR USE FOR PREVENTING AND/OR TREATING A DISEASE LINKED WITH CEREBRAL HYPOPERFUSION

#1750
20230015276
2023-01-19

METHODS AND COMPOSITIONS TO INCREASE SOMATIC CELL NUCLEAR TRANSFER (SCNT) EFFICIENCY BY REMOVING HISTONE H3-LYSINE TRIMETHYLATION

#1751
20230013636
2023-01-19

EXOSOMES-BASED THERAPY FOR LIVER FIBROSIS AND OTHER DISEASES WITH FIBROSIS

#1752
20230013224
2023-01-19

RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use

#1753
20230012420
2023-01-12

METHODS AND COMPOSTIONS FOR INHIBITING P97

#1754
20230011179
2023-01-12

NUCLEOSIDE DERIVATIVE AND USE THEREOF

#1755
20230010683
2023-01-12

TISSUE FOR USE AS ALLOGENEIC OR XENOGENEIC TRANSPLANT AND METHOD FOR ITS PRODUCTION

#1756
20230010288
2023-01-12

RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES

#1757
20230009757
2023-01-12

COMBINATION THERAPY FOR C3 INHIBITION

#1758
20230002775
2023-01-05

METHOD OF TREATING CANCER AND METHOD OF SENSITIZING CANCER CELLS TO THE ACTION OF CHEMOTHERAPEUTIC AGENTS VIA GROWTH HORMONE RECEPTOR ANTAGONISTS OR KNOCK DOWN

#1759
20230002774
2023-01-05

METHODS AND COMPOSTIONS FOR INHIBITING CORONAVIRAL REPLICATION

#1760
20230002773
2023-01-05

RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use

#1761
20230002772
2023-01-05

PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1762
20230002771
2023-01-05

Compounds and methods for modulating factor XII

#1763
20230002770
2023-01-05

IL-34 ANTISENSE AGENTS AND METHODS OF USING SAME

#1764
20230002768
2023-01-05

Compositions and methods for inhibiting gene expression of alpha-1 antitrypsin

#1765
20230002767
2023-01-05

RNAi Agents for Inhibiting Expression of Mucin 5AC (MUC5AC), Compositions Thereof, and Methods of Use

#1766
20230002766
2023-01-05

CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY

#1767
20230002754
2023-01-05

Vitro Cleavage of DNA Using Argonaute

#1768
20230001020
2023-01-05

SELECTIVE EXPANSION OF GENE-TARGETED CELLS

#1769
20230001002
2023-01-05

Muscle targeting complexes and uses thereof for treating dystrophinopathies

#1770
20230000999
2023-01-05

COMPOSITIONS AND METHODS FOR NUCLEIC ACID DELIVERY

#1771
20220411870
2022-12-29

Treatment Of Obesity With G-Protein Coupled Receptor 75 (GPR75) Inhibitors

#1772
20220411823
2022-12-29

PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF

#1773
20220411817
2022-12-29

METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION

#1774
20220411802
2022-12-29

METHODS OF CANCER TREATMENT BY DELIVERY OF siRNAs AGAINST NSD3

#1775
20220411801
2022-12-29

XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1776
20220411800
2022-12-29

RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE

#1777
20220411798
2022-12-29

Hippo and dystrophin complex signaling in cardiomyocyte renewal

#1778
20220411797
2022-12-29

Twist signaling inhibitor compositions and methods of using the same

#1779
20220411792
2022-12-29

NUCLEIC ACID COMPOSITIONS

#1780
20220409735
2022-12-29

Compositions and methods of treating muscle dystrophy

#1781
20220409663
2022-12-29

ENGINEERED T CELLS AND TUMOR-INFILTRATING LYMPHOCYTES TO OVERCOME IMMUNOSUPPRESSION IN THE TUMOR MICROENVIRONMENT

#1782
20220408732
2022-12-29

Control of plant pests using RNA molecules

#1783
20220403395
2022-12-22

COMPOSITION FOR INHIBITING GROWTH OF CANCER STEM CELLS, CONTAINING WDR34 INHIBITOR, AND USE THEREOF

#1784
20220403382
2022-12-22

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#1785
20220403381
2022-12-22

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#1786
20220403377
2022-12-22

MODIFIED iRNA AGENTS

#1787
20220403356
2022-12-22

3' UTR CRISPR-DCAS 13 ENGINEERING SYSTEM AND METHODS OF USING SAME

#1788
20220403021
2022-12-22

Targeting Synaptogyrin-3 in Tauopathy Treatment

#1789
20220402947
2022-12-22

Trialkyne linking agents and methods of use

#1790
20220396799
2022-12-15

THERAPEUTIC INHIBITION OF LACTATE DEHYDROGENASE AND AGENTS THEREFOR

#1791
20220396793
2022-12-15

Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA

#1792
20220396791
2022-12-15

RNAi Agents for Inhibiting Expression of Receptor for Advanced Glycation End-products, Compositions Thereof, and Methods of Use

#1793
20220395540
2022-12-15

TREATMENT OF COVID-19 LUNG INJURY USING UMBILICAL CORD PLASMA BASED COMPOSITIONS

#1794
20220389430
2022-12-08

CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT

#1795
20220389429
2022-12-08

COMPOSITIONS AND METHODS FOR SILENCING UGT1A1 GENE EXPRESSION

#1796
20220389428
2022-12-08

Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof

#1797
20220389424
2022-12-08

Modified double-stranded RNA agents

#1798
20220389390
2022-12-08

Compositions and methods of treatment

#1799
20220387612
2022-12-08

Compositions and methods for transport across the blood brain barrier

#1800
20220387600
2022-12-08

CONJUGATES AND METHODS FOR TREATING LIVER FIBROSIS