109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
Selective inhibition of T follicular helper cells for treatment of autoimmune disorders
#1502METHODS AND COMPOSITIONS OF RNA NANOSTRUCTURES FOR REPLICATION AND SUB-GENOMIC EXPRESSION BY RNA-DIRECTED RNA POLYMERASE
#1503COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#1504LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS
#1505METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS
#1506METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS
#1507COMPOSITIONS AND METHODS FOR INHIBITING NUCLEAR RECEPTOR SUBFAMILY 1 GROUP H MEMBER 3 (NR1H3) EXPRESSION
#1508Transmembrane protease, serine 6 (TMPRSS6) iRNA compositions and methods of use thereof
#1509METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#1510CILP-1 Inhibitors for Use in the Treatment of Dilated Cardiomyopathies
#1511MULTIMERIC OLIGONUCLEOTIDES WITH DIVIDED STRANDS
#1512D-SERINE TRANSPORT MODIFIER AND SCREENING METHOD THEREOF, AND SCREENING METHOD OF D-SERINE TRANSPORTER PROTEIN
#1513OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#1514GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY
#1515METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA DIRECTED MODULATION OF TRANSCRIPTION
#1516Cellular Ablation of HLA-Class I MHC
#1517MEDICAMENT USED FOR TREATING CHOLANGIOCARCINOMA WITH KRAS MUTATIONS
#1518COMPOSITIONS AND METHODS OF INDUCING RNAI OR TYPE I IFN COMPETENT CELLS AND USES THEREOF
#1519COMPOSITIONS AND METHODS FOR TREATING HYPERTRIGLYCERIDEMIA
#1520MAPT RNA INTERFERENCE AGENTS
#1521EDIBLE PLANT EXOSOME-LIKE NANOVECTORS FOR VACCINATION
#1522NUCLEIC ACID MOLECULES FOR REDUCTION OF PAPD5 OR PAPD7 MRNA FOR TREATING HEPATITIS B INFECTION
#1523RNAi FOR CONTROL OF PHLOEM SAP-FEEDING INSECTS IN CROP PLANTS
#1524GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS
#1525SYSTEMS AND METHODS FOR TREATING LEVODOPA DYSKINESIA, ENHANCING MOTOR BENEFIT, AND DELAYING DISEASE PROGRESSION
#1526DYNAMIN 2 INHIBITOR FOR THE TREATMENT OF CENTRONUCLEAR MYOPATHIES
#1527FIDGETIN-LIKE 2 AS A TARGET TO ENHANCE SKIN GRAFT HEALING
#1528AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#1529Biomarkers Related to Oral Squamous Cell Carcinoma and Methods of Diagnosis and Treatment Thereof
#1530DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR TREATING COVID-19 CONTAINING SAME
#1531UTILIZING RNA INTERFERENCE AGAINST SARS-COV-2
#1532COMPOSITIONS AND METHODS FOR CONTROLLING LEPTINOTARSA
#1533EXOSOME-DERIVED PIWI-INTERACTING RNA AND METHODS OF USE THEREOF
#1534MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1535DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#1536MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR MODULATION OF GENES ASSOCIATED WITH MUSCLE HEALTH
#1537PREPARATION METHOD OF ARTIFICIAL ANTIBODY
#1538MULTI-CONJUGATES COMPRISING MULTIPLE LIGANDS
#1539SYNTHESIS OF 3'N NUCLEOSIDES THROUGH OXIME INTERMEDIATES AND RELATED COMPOUNDS
#1540Compositions and methods of treating muscle atrophy and myotonic dystrophy
#1541Compositions and methods of treating muscle atrophy and myotonic dystrophy
#1542LINKER COMPOUNDS
#1543MODULATORS OF FOXP3 EXPRESSION
#1544TRANSMEMBRANE SERINE PROTEASE 2 (TMPRSS2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1545COMPOSITION FOR PREVENTING OR TREATING DISEASE CAUSED BY MUSCLE LOSS, COMPRISING AGENT INHIBITING PHF20
#1546OLIGONUCLEOTIDES FOR SOD1 MODULATION
#1547MULTI-TARGETED siRNA FOR TREATING CANCERS
#1548NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#1549Composition of drug targets and method of using thereof
#1550APOLIPOPROTEIN E (APOE) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1551CARDIAC CELL PROLIFERATION BY ADMINISTERING INHIBITORS OF SAV1, NF2, MOB1 AND/OR MUTANT SRF
#1552COMPOUNDS AND METHODS FOR THE TREATMENT OF CANCER
#1553METHODS FOR THE DIAGNOSIS AND TREATMENT OF CYTOKINE RELEASE SYNDROME
#1554Human antibodies to the human glucagon receptor (HGCGR) and methods of use thereof to lower blood glucose or ketone levels
#1555RECOMBINANT POLYPEPTIDES FOR MEMBRANE FUSION AND USES THEREOF
#1556Treating metastatic cancer and model systems for metastatic disease
#1557METHODS FOR TREATING GAIN-OF-FUNCTION DISORDERS COMBINING GENE EDITING AND GENE THERAPY
#1558COMPOSITIONS AND METHODS FOR THE TREATMENT OF A BETA-CATENIN-ASSOCIATED DISEASE OR DISORDER
#1559COMPOSITIONS AND METHODS FOR FUNGAL INHIBITION USING MINICELL-BASED RNAi
#1560COMPOSITIONS FOR TRANSFER OF CARGO TO CELLS
#1561COMPOSITIONS AND METHODS FOR INHIBITING MARC1 GENE EXPRESSION
#1562PRODUCTS FOR SUPPRESSING OR REDUCING THE EXPRESSION OR ACTIVITY OF A SNORNA AND USES THEREOF IN THE TREATMENT OF CANCER
#1563Modified double-stranded RNA agents
#1564COMPOSITIONS AND METHODS FOR THE DELIVERY OF AGENTS TO BIOLOGICAL TARGETS
#1565COMPOSITIONS AND METHODS FOR TREATING NEOPLASIA
#1566Hybridosomes, compositions comprising the same, processes for their production and uses thereof
#1567IMMUNOLOGICALLY COMPATIBLE AND REVERSIBLE UNIVERSAL PLURIPOTENT STEM CELL AND APPLICATION THEREOF
#1568METHODS FOR INDUCING BILE ACID SULFOTRANSFERASE SULT2A FOR TREATING METABOLIC DISORDERS
#1569Medication and diagnostic kit for inhibiting metastasis and invasion of breast cancer, shRNA molecule for silencing expression of human LINC01614 and application thereof
#1570METHODS AND COMPOSITIONS FOR MODULATING GENE EXPRESSION
#1571TARGETED ANTIVIRAL DRUGS
#1572DEPLETION OF EXT1 EXPRESSION AND/OR ACTIVITY IMPROVES CELLULAR PRODUCTION OF BIOLOGICAL ENTITIES
#1573COMPOUNDS AND METHODS FOR REDUCING PSD3 EXPRESSION
#1574COMPOSITIONS AND METHODS FOR INTRANASAL TREATMENT WITH DOUBLE STRANDED RNA
#1575METHOD OF STIMULATING PROLIFERATION OF A CELL
#1576COMPOSITIONS AND METHODS FOR SILENCING SCN9A EXPRESSION
#1577TARGETING THE PALMOTYLATION/DEPALMOTYLATION CYCLE TO TREAT INFLAMMATORY DISEASES
#1578MODIFIED SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF
#1579USE OF LNCRNA XR_595534.2 IN PREPARATION OF MEDICINE FOR TREATMENT OR PREVENTION OF CHRONIC PAIN
#1580Composition for preventing or treating diseases caused by overexpression of chemokine CXCL1, containing death receptor inhibitor as active ingredient
#1581EXPRESSION OF FC-CONTAINING PROTEINS
#1582COMPOUND COMPRISING A NUCLEIC ACID AND A HALF-LIFE EXTENSION MOTIF
#1583Prekallikrein-modulating compositions and methods of use thereof
#1584METHODS AND COMPOSITIONS FOR APTAMER-DRIVEN SURFACE FORMULATION OF SELF-FORMING POLYNUCLEOTIDE NANOPARTICLES
#1585COMPOSITIONS AND METHODS FOR INHIBITING TDP-43 AND FUS AGGREGATION
#1586EXTRACELLULAR VESICLE SECRETION REDUCING AGENT FOR REDUCING EXTRACELLULAR VESICLE SECRETION, AND USE OF THE SAME
#1587MODIFIED SHORT-INTERFERING RNA COMPOSITIONS AND THEIR USE IN THE TREATMENT OF CANCER
#1588ARTC1 LIGANDS FOR CANCER TREATMENT
#1589COMPOSITIONS AND METHODS OF MODULATING B CELL RESPONSE
#1590TREATMENT OF ALT CANCERS
#1591METHODS FOR ENHANCING VASCULAR DENSITY
#1592DESIGN METHOD FOR OPTIMIZED RIG-I LIGANDS
#1593MULTIMERIC OLIGONUCLEOTIDES WITH DIVIDED STRANDS
#1594TREATMENT OF COVID-19 WITH REVERSE MICELLE SYSTEM COMPRISING UNMODIFIED OLIGONUCLEOTIDES
#1595SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY
#1596METHOD FOR TREATING CARDIOVASCULAR DISEASE
#1597METHODS AND COMPOSITIONS FOR INACTIVATING INTERLEUKIN-2-INDUCIBLE T-CELL KINASE (ITK)
#1598SiRNA molecule inhibiting the expression of the PCSK9 gene and use thereof
#1599RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#16001'-ALKYL MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE
#1601ALPHA-2A ADRENERGIC RECEPTOR (ADRA2A) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1602GENE SILENCING AGENTS FOR TARGETING CORONAVIRUS GENES AND USES THEREOF
#1603COMPOSITIONS AND METHODS FOR SILENCING VEGF-A EXPRESSION
#1604PRODUCTS AND COMPOSITIONS
#1605ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1606DOUBLE-STRANDED OLIGONUCLEOTIDE, COMPOSITION AND CONJUGATE COMPRISING DOUBLE-STRANDED OLIGONUCLEOTIDE, PREPARATION METHOD THEREOF AND USE THEREOF
#1607USE OF CDON INHIBITORS FOR THE TREATMENT OF ENDOTHELIAL DYSFUNCTION
#1608METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1
#1609TREATMENT OF COVID-19 WITH REVERSE MICELLE SYSTEM COMPRISING UNMODIFIED OLIGONUCLEOTIDES
#1610Fc FRAGMENT OF IgG RECEPTOR AND TRANSPORTER (FCGRT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1611LEUCINE-RICH REPEAT KINASE 2 (LRRK2) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1612MANNAN BINDING LECTIN SERINE PEPTIDASE 2 (MASP2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1613RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#1614Composition for preventing or treating keloids or hypertrophic scars
#16154'-O-METHYLENE PHOSPHONATE NUCLEIC ACIDS AND ANALOGUES THEREOF
#1616RNA-DIRECTED DNA CLEAVAGE BY THE Cas9-crRNA COMPLEX
#1617Deaminase-based RNA sensors
#1618ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1619METHODS AND COMPOSITIONS FOR TREATMENT OF ATHEROSCLEROSIS
#1620USP10 TARGETED SELF-DELIVERABLE SIRNA COMPOSITIONS AND METHODS FOR PREVENTING OR INHIBITING FIBROSIS AND/OR SCARRING
#1621USE OF COPS3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#1622CHIRALLY-ENRICHED DOUBLE-STRANDED RNA AGENTS
#1623COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#1624Immunomodulatory RNA
#1625DIAGNOSTIC METHODS USING PCG-1A EXPRESSION
#1626HYPERBRANCHED POLYMERS AND POLYPLEXES AND DNA OR RNA DELIVERY SYSTEMS INCLUDING THE SAME
#1627USE OF SARAF INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#1628RNAI INDUCED HUNTINGTIN GENE SUPPRESSION
#1629Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
#1630USE OF SCAMP3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#1631MUSCLE-TARGETING COMPLEXES AND USES THEREOF IN TREATING MUSCLE ATROPHY
#1632NANOPARTICLES FOR EXPRESSION OF GENES OF INTEREST AND/OR REGULATION OF SIGNALING PATHWAYS
#1633HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1634SYNTHETIC PROCESSES AND INTERMEDIATES
#1635Methods Of Treating Clonal Hematopoiesis Of Indeterminate Potential (CHIP) With Lymphocyte Antigen 75 (LY75), Cluster Of Differentiation 164 (CD164), Or Poly(ADP-Ribose) Polymerase 1 (PARP1) Inhibitors
#1636METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF KRAS BY ASYMMETRIC DOUBLE-STRANDED RNA
#1637MODIFIED DOUBLE-STRANDED RNA AGENTS
#1638Targeted compositions
#1639Compound and application thereof
#1640TRIALKYL CATIONIC LIPIDS AND METHODS OF USE THEREOF
#1641METHODS FOR REDUCING HTT EXPRESSION
#1642COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-1 ANTITRYPSIN EXPRESSION
#1643POLY(BETA-AMINO ESTER)-CO-POLYETHYLENE GLYCOL (PEG-PBAE-PEG) POLYMERS FOR GENE AND DRUG DELIVERY
#1644Methods Of Treating Chronic Kidney Disease (CKD) With Inhibitors Of Protective Loss-Of-Function Genes
#1645METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER
#1646OVERLAPPING THERAPEUTIC STRATEGIES FOR CYSTINOSIS TREATMENT AND COSMETIC SKIN DARKENING
#1647KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1648Increasing gene expression
#1649Compositions comprising reversibly modified oligonucleotides and uses thereof
#1650Cancer treatment using siRNA to modulate expression of PRDM2/RIZ protein
#1651Treatment Of Glaucoma With Rho Guanine Nucleotide Exchange Factor 12 (ARHGEF12) Inhibitors
#1652SERINE PROTEASE INHIBITORS FOR SUPPRESSING OR PREVENTING ANAPHYLACTIC REACTION
#1653VITAMIN B6-COUPLED POLYOL-BASED POLYDIXYLITOL GENE TRANSPORTER COMPRISING PEPTIDE BINDING SPECIFICALLY TO CANCER STEM CELL AND CANCER STEM CELL-TARGETED THERAPY TECHNIQUE
#1654ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS
#1655STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1656Compositions and methods for delivery of nucleic acids to cells
#1657Methods of treating cancers having a BRCA1 and/or BRCA2 mutation(s)
#1658COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSING OF METHYLATION-CONTROLLED J-PROTEIN (MCJ)
#1659PRODUCTS AND COMPOSITIONS
#1660CHEMICALLY MODIFIED OLIGONUCLEOTIDES WITH IMPROVED SYSTEMIC DELIVERY
#1661Targeted therapy composition and its use for suppressing breast cancer cell proliferation, migration or invasion
#1662TOPICAL DELIVERY OF RNA INTERFERENCE AGENTS USING IONIC LIQUID
#1663Compositions and methods for delivery of nucleic acids to cells
#1664Adeno-associated virus for activating RNA-NEAT1 over-expression and applications thereof
#1665DRUG FOR CURATIVE THERAPY OF INTRACTABLE HEREDITARY RENAL ALPORT SYNDROME
#1666ANTICANCER ADJUVANT AND PHARMACEUTICAL COMPOSITION FOR TREATING ANTICANCER-AGENT-RESISTANT CANCER, AND KIT COMPRISING SAME
#1667METHODS AND MATERIALS FOR TREATING CANCER
#1668Methods and compositions for reducing pathogenic isoforms
#1669COMPOSITIONS COMPRISING BACTERIALLY DERIVED MINICELLS AND METHODS OF USING THE SAME
#1670RNAi CONSTRUCTS AND METHODS FOR INHIBITING LPA EXPRESSION
#1671COMPOSITIONS AND METHODS FOR TREATING OR AMELIORATING A MYCOBACTERIUM TUBERCULOSIS INFECTION
#1672Composition for preventing or treating cognitive dysfunction including inhibitor or MECP2 expression
#1673VECTORIZED ANTIBODIES (vAb) AND USES THEREOF
#1674Treatment Of Inflammatory Diseases With RAS Protein Activator Like 3 (RASAL3) Inhibitors
#1675TREATMENT OF THYMIC STROMAL LYMPHOPOIETIN (TSLP) RELATED DISEASES BY INHIBITION OF LONG-FORM TSLP TRANSCRIPTS
#1676THERAPY OF RAS-DEPENDENT CANCERS
#1677REPROGRAMMING THE METABOLOME TO DELAY ONSET OR TREAT NEURODEGENERATION
#1678Multi-conjugate of siRNA and preparing method thereof
#1679METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF ALPHA-1 ANTITRYPSIN BY DOUBLE-STRANDED RNA
#1680APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1681Methods and compositions for genomic integration
#1682METHODS AND COMPOSITIONS FOR INDUCING APOPTOSIS IN CANCER STEM CELLS
#1683ANTAGONISM AS A THERAPY FOR TDP-43 PROTEINOPATHIES
#1684METHODS AND USES FOR PROPROTEIN CONVERTASE SUBTILISIN KEXIN 9 (PCSK9) INHIBITORS
#1685TARGETED AND LOCALIZED IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#16864′-phosphate analogs and oligonucleotides comprising the same
#1687RIBONUCLEOPROTEINS FOR RNA THERAPEUTICS DELIVERY AND GENE SILENCING
#1688FORMULATIONS FOR DELIVERY OF OLIGONUCLEOTIDES TO LUNG CELLS
#1689Modulation Of Endoplasmic Reticulum Aminopeptidase 2 (ERAP2)-Mediated Immune Response
#1690Methods and compositions for the specific inhibition of transthyretin (TTR) by double-stranded RNA
#1691INHIBITION OF TAP63 REGULATED ONCOGENIC LONG NON-CODING RNAS (TROLLS) IN THE TREATMENT OF CANCER
#1692METHODS AND COMPOSITIONS FOR THE INHIBITION OF HEPATITIS B AND HEPATITIS D VIRUS INFECTIONS
#1693ATAXIN3 (ATXN3) RNAI AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1694NOVEL PRECURSOR MIRNA AND APPLICATION THEREOF IN TUMOR TREATMENT
#1695Methods of treating decreased bone mineral density with cluster of differentiation 109 (CD109) inhibitors
#1696COMPOUNDS AND METHODS FOR REDUCING APP EXPRESSION
#1697INHIBITION OF DENND5B EXPRESSION FOR TREATING HEPATIC STEATOSIS
#1698METHODS AND COMPOSITIONS FOR MODULATING GENE EXPRESSION
#1699COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
#1700USE OF POTASSIUM CHANNEL INHIBITOR FOR TREATING DEPRESSION
#1701MODIFIED DOUBLE STRANDED OLIGONUCLEOTIDE
#1702PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF
#1703COMPOSITIONS AND METHODS OF TREATMENT FOR LYTIC AND LYSOGENIC VIRUSES
#1704COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#1705siRNA based on RNA sequence of SARS-CoV-2 and use thereof
#1706System for the biocontrol of white spot syndrome virus (WSSV) in aquaculture
#1707TREATMENT OF PROGRESSIVE SUPRANUCLEAR PALSY
#1708Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy
#1709METHODS AND COMPOSITIONS FOR TREATING ATHEROSCLEROSIS
#1710CTGF GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE, AND A COMPOSITION FOR PREVENTING AND TREATING FIBROTIC DISEASES AND RESPIRATORY-RELATED DISEASES COMPRISING SAME
#1711Compositions and methods for inhibiting mitochondria amidoxime reducing component 1 (MARC1) expression
#1712ADOPTIVE CELL THERAPY WITH ZBTB20 SUPPRESSION
#1713Methods and Compositions for Modulationg Heterochromatin Dysfunction, Genomic Instability, and Associate Conditions
#1714METHOD FOR TREATING ANGELMAN SYNDROME AND RELATED DISORDERS
#1715COMPOSITIONS AND METHODS FOR SILENCING DNAJB1-PRKACA FUSION GENE EXPRESSION
#1716PERICYTE-SPARING THERAPY
#1717PROCESS FOR BUILDING NANOPARTICLE-BASED DRUG CARRIERS VIA PROTEIN CORONA MODULATION
#1718Modified EC7 Cells Having Low Toxicity to Viral Production Payloads
#1719INHIBITORS OF KDM5A FOR USE IN TREATMENT OF IDIOPATHIC INFLAMMATORY MYOPATHIES
#1720Treatment Of Psoriasis With Interferon Induced Helicase C Domain 1 (IFIH1) Inhibitors
#1721ENGINEERED IMMUNE CELLS WITH REDUCED TOXICITY AND USES THEREOF
#1722Compositions and methods for treating cancer
#1723Targeting cell tropism receptors to inhibit cytomegalovirus infection
#1724Treatment Of Cognitive Impairment With Alpha-N-Acetylgalactosaminide Alpha-2,6-Sialyltransferase 5 (ST6GALNAC5) Inhibitors
#1725Compositions and methods for delivery of nucleic acids to cells
#1726HSD17B13 VARIANTS AND USES THEREOF
#1727TARGETING GLIOBLASTOMA STEM CELLS THROUGH THE TLX-TET3 AXIS
#1728RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#1729METHODS AND COMPOSITIONS TO PROMOTING RETINAL REGENERATION USING PROX1 MIGRATION INHIBITOR AS ACTIVE INGREDIENT
#1730Tunable Reversir™ compounds
#1731MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#1732APOLIPOPROTEIN B ANTAGONIST
#1733Treatment of Hypertension With Solute Carrier Family 9 Isoform A3 Regulatory Factor 2 (SLC9A3R2) Inhibitors
#1734COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#1735Inhibitors of Cancer Biomarkers and Uses Thereof
#1736Compositions and methods for organ specific delivery of nucleic acids
#1737Compounds and methods for reducing IFNAR1 expression
#1738Nucleic acids for inhibiting expression of C3 in a cell
#1739NEUROFILAMENT LIGHT CHAIN (NFL) AS A BIOMARKER FOR TRANSTHYRETIN AMYLOIDOSIS POLYNEUROPATHY
#1740NOVEL RNA THERAPEUTICS AND USES THEREOF
#1741Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#1742USE OF GP73 INHIBITOR IN PREPARATION OF MEDICINE FOR TREATING DIABETES
#1743Methods Of Treating Decreased Bone Mineral Density With Kringle Containing Transmembrane Protein 1 (KREMEN1) Inhibitors
#1744Oligonucleotides for SARS-CoV-2 modulation
#1745Methods for reactivating genes on the inactive X chromosome
#1746COMPOUNDS AND METHODS FOR MODULATING C90RF72
#1747Nucleic acids for inhibiting expression of PROS1 in a cell
#1748INHIBITING THE RNA METHYLTRANSFERASE METTL3 OR ITS INTERACTION WITH EIF3H TO SUPPRESS ONCOGENE TRANSLATION AND TUMORIGENESIS
#1749AN UBIQUITIN LIGASE INHIBITOR FOR USE FOR PREVENTING AND/OR TREATING A DISEASE LINKED WITH CEREBRAL HYPOPERFUSION
#1750METHODS AND COMPOSITIONS TO INCREASE SOMATIC CELL NUCLEAR TRANSFER (SCNT) EFFICIENCY BY REMOVING HISTONE H3-LYSINE TRIMETHYLATION
#1751EXOSOMES-BASED THERAPY FOR LIVER FIBROSIS AND OTHER DISEASES WITH FIBROSIS
#1752RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#1753METHODS AND COMPOSTIONS FOR INHIBITING P97
#1754NUCLEOSIDE DERIVATIVE AND USE THEREOF
#1755TISSUE FOR USE AS ALLOGENEIC OR XENOGENEIC TRANSPLANT AND METHOD FOR ITS PRODUCTION
#1756RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#1757COMBINATION THERAPY FOR C3 INHIBITION
#1758METHOD OF TREATING CANCER AND METHOD OF SENSITIZING CANCER CELLS TO THE ACTION OF CHEMOTHERAPEUTIC AGENTS VIA GROWTH HORMONE RECEPTOR ANTAGONISTS OR KNOCK DOWN
#1759METHODS AND COMPOSTIONS FOR INHIBITING CORONAVIRAL REPLICATION
#1760RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#1761PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1762Compounds and methods for modulating factor XII
#1763IL-34 ANTISENSE AGENTS AND METHODS OF USING SAME
#1764Compositions and methods for inhibiting gene expression of alpha-1 antitrypsin
#1765RNAi Agents for Inhibiting Expression of Mucin 5AC (MUC5AC), Compositions Thereof, and Methods of Use
#1766CHEMICALLY MODIFIED OLIGONUCLEOTIDES TARGETING BROMODOMAIN CONTAINING PROTEIN 4 (BRD4) FOR IMMUNOTHERAPY
#1767Vitro Cleavage of DNA Using Argonaute
#1768SELECTIVE EXPANSION OF GENE-TARGETED CELLS
#1769Muscle targeting complexes and uses thereof for treating dystrophinopathies
#1770COMPOSITIONS AND METHODS FOR NUCLEIC ACID DELIVERY
#1771Treatment Of Obesity With G-Protein Coupled Receptor 75 (GPR75) Inhibitors
#1772PLATELETS TRANSFECTED BY EXOGENOUS GENETIC MATERIAL AND PLATELET MICROPARTICLES OBTAINED BY SAID TRANSFECTED PLATELETS, METHOD FOR THE PREPARATION AND USES THEREOF
#1773METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#1774METHODS OF CANCER TREATMENT BY DELIVERY OF siRNAs AGAINST NSD3
#1775XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1776RNA MOLECULE, CHIMERIC NA MOLECULE, DOUBLE-STRANDED RNA MOLECULE, AND DOUBLE-STRANDED CHIMERIC NA MOLECULE
#1777Hippo and dystrophin complex signaling in cardiomyocyte renewal
#1778Twist signaling inhibitor compositions and methods of using the same
#1779NUCLEIC ACID COMPOSITIONS
#1780Compositions and methods of treating muscle dystrophy
#1781ENGINEERED T CELLS AND TUMOR-INFILTRATING LYMPHOCYTES TO OVERCOME IMMUNOSUPPRESSION IN THE TUMOR MICROENVIRONMENT
#1782Control of plant pests using RNA molecules
#1783COMPOSITION FOR INHIBITING GROWTH OF CANCER STEM CELLS, CONTAINING WDR34 INHIBITOR, AND USE THEREOF
#1784COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#1785COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1786MODIFIED iRNA AGENTS
#17873' UTR CRISPR-DCAS 13 ENGINEERING SYSTEM AND METHODS OF USING SAME
#1788Targeting Synaptogyrin-3 in Tauopathy Treatment
#1789Trialkyne linking agents and methods of use
#1790THERAPEUTIC INHIBITION OF LACTATE DEHYDROGENASE AND AGENTS THEREFOR
#1791Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA
#1792RNAi Agents for Inhibiting Expression of Receptor for Advanced Glycation End-products, Compositions Thereof, and Methods of Use
#1793TREATMENT OF COVID-19 LUNG INJURY USING UMBILICAL CORD PLASMA BASED COMPOSITIONS
#1794CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT
#1795COMPOSITIONS AND METHODS FOR SILENCING UGT1A1 GENE EXPRESSION
#1796Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof
#1797Modified double-stranded RNA agents
#1798Compositions and methods of treatment
#1799Compositions and methods for transport across the blood brain barrier
#1800CONJUGATES AND METHODS FOR TREATING LIVER FIBROSIS