109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
Compositions and methods for organ specific delivery of nucleic acids
#1802Organic compositions to treat HSF1-related diseases
#1803ASYMMETRIC SIRNA INHIBITING EXPRESSION OF PD-1
#1804COMPOUNDS AND METHODS FOR REDUCING APP EXPRESSION
#1805RNA interference mediated inhibition of prolyl hydroxylase domain 2 (PHD2) gene expression using short interfering nucleic acid (siNA)
#1806Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof
#1807SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF FOR CORONAVIRUS DISEASES
#1808TARGETING NONSENSE-MEDIATED DECAY TO ACTIVATE P53 PATHWAY FOR THE TREATMENT OF CANCER
#1809MOLECULAR GUIDE SYSTEM PEPTIDES AND USES THEREOF
#1810NUCLEIC ACID DELIVERY ENHANCER
#1811HUNTINGTIN (HTT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#1812ORAL DELIVERY OF OLIGONUCLEOTIDES
#1813GENE THERAPY TARGETING COCHLEAR CELLS
#1814Nucleus-encoded male sterility through mutation in cytochrome P450 oxidase
#1815Temperature-based transient delivery of nucleic acids and proteins to cells and tissues
#1816siRNA EXPRESSION VECTOR
#1817VECTOR SYSTEM FOR EXPRESSING REGULATORY RNA
#1818TREATMENT OF RENAL CYSTIC DISEASE
#1819REACTIVATING P53 MUTANTS FOR CANCER TREATMENT BY TARGETING PROLIDASE (PEPD)
#1820METHODS OF CANCER TREATMENT BY INHIBITION OF VASCULOGENESIS AND GLI1
#1821COMPOSITIONS AND METHODS FOR LOADING EXTRACELLULAR VESICLES WITH CHEMICAL AND BIOLOGICAL AGENTS/MOLECULES
#1822Dynamic pharmacokinetic-modifying anchors
#1823ANTISENSE COMPOUNDS AND USES THEREOF
#1824COMPOSITIONS CONTAINING NUCLEIC ACID NANOPARTICLES WITH MODULAR FUNCTIONALITY
#1825FN3 domain-siRNA conjugates and uses thereof
#1826TREATMENT/PREVENTION OF DISEASE BY LINC COMPLEX INHIBITION
#1827BIODEGRADABLE LIPIDS FOR THE DELIVERY OF ACTIVE AGENTS
#1828THREE-DIMENSIONAL FLOW PATH STRUCTURE BODY AND NANOPARTICLE PRODUCTION METHOD USING SAME
#1829METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#1830OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS
#1831Methods of treating liver diseases with phosphodiesterase 3B (PDE3B) inhibitors
#1832RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#1833Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#1834Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#1835METHOD OF STIMULATING PROLIFERATION OF A CELL
#1836Method for promoting differentiation of pluripotent stem cells by reducing undifferentiated state thereof
#1837COMPOSITIONS AND METHODS FOR TREATING CYTOTOXIC T CELL RESISTANT TUMORS
#1838CD5 SPECIFIC T CELL RECEPTOR CELL OR GENE THERAPY
#1839TREATMENT OF MAJOR DEPRESSIVE DISORDER BY LOW DOSE INTERLEUKIN-2
#1840INSECT EXTRACELLULAR VESICLES FOR DELIVERY OF NUCLEIC ACIDS
#1841Superoxide dismutase 1 (SOD1) iRNA compositions and methods of use thereof for treating or preventing superoxide dismutase 1-(SOD1-) associated neurodegenerative diseases
#1842NUCLEIC ACID, COMPOSITION AND CONJUGATE COMPRISING THE SAME, PREPARATION METHOD AND USE THEREOF
#1843METHODS AND COMPOSITIONS FOR TYPE 2 DIABETES THERAPY
#1844Enhancing Production of Lentiviral Vectors
#1845PHARMACEUTICAL COMPOSITION CONTAINING HERES EXPRESSION INHIBITOR FOR PREVENTING OR TREATING SQUAMOUS CELL CARCINOMA
#1846PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1847p63 inactivation for the treatment of heart failure
#1848LNCRNAS FOR THERAPY AND DIAGNOSIS OF CARDIAC HYPERTROPHY
#1849HYBRID NUCLEIC ACID MOLECULES AND THEIR USE
#1850GNAQ targeted dsRNA compositions and methods for inhibiting expression
#1851Oligonucleotide-ligand conjugates and process for their preparation
#1852Enhanced immune cells using dual shRNA and composition including the same
#1853CD25 PRE-SELECTIVE COMBINATION ANTI-HIV VECTORS, TARGETING VECTORS, AND METHODS OF USE
#1854Exosome-Mediated Transfection for Delivery of Nucleic Acids
#1855RNAi insecticide materials and methods
#1856Compositions and methods for inhibiting nuclear receptor subfamily 1 group H member 3 (NR1H3) expression
#1857RNAI CONSTRUCTS FOR INHIBITING SLC30A8 EXPRESSION AND METHODS OF USE THEREOF
#1858SUGAR CHAIN-RELATED GENE AND USE THEREOF
#1859COMPOSITIONS AND METHODS FOR INHIBITING KETOHEXOKINASE (KHK)
#1860METHODS FOR DEPLETION OF DELETERIOUS MITOCHONDRIAL GENOMES
#1861OLIGONUCLEOTIDES FOR TREATMENT OF ANGIOPOIETIN LIKE 4 (ANGPTL4) RELATED DISEASES
#1862Methods for treating SARS-CoV-2 infection
#1863INHIBITOR AGAINST EXPRESSION OF IMMUNE CHECKPOINT MOLECULE
#1864USE OF REAGENT FOR DOWN-REGULATING CIRCULAR GENE EXPRESSION IN PREPARATION OF DRUGS FOR PREVENTING AND/OR TREATING PULMONARY FIBROSIS AND DRUG THEREOF
#1865TREATMENT OF HR DEFICIENT CANCER
#1866METHODS OF TREATING OR SELECTING A TREATMENT FOR A SUBJECT RESISTANT TO TNF INHIBITOR USING A NLRP3 ANTAGONIST
#1867PARTICLES AND COMPOSITIONS COMPRISING THE SAME FOR TRANSFECTION
#1868MELANOGENESIS DETECTION METHOD USING FAM86A
#1869Products and methods for inhibition of expression of dynamin-1 variants
#1870SiRNA, medical compositions, and methods for treating type ii diabetes using the same
#1871VASCULOGENIC FIBROBLASTS
#1872TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#1873INHIBITION OF MTHFD1L FOR USE IN HYPERTROPHIC HEART DISEASE AND HEART FAILURE
#1874COMPOSITIONS AND METHODS FOR TREATMENT AND PREVENTION OF ALZHEIMER'S DISEASE
#1875HERV INHIBITORS FOR USE IN TREATING TAUOPATHIES
#1876CD71 binding fibronectin type III domains
#1877ANTIBODY-BIOMOLECULE CONJUGATES LINKED THROUGH MULTIFUNCTIONAL MACROMOLECULE AND USES THEREOF
#1878Tumor-Targeting Polypeptide Nanoparticle Delivery System for Nucleic Acid Therapeutics
#1879METHODS OF TREATING CANCER USING TIGIT INHIBITORS AND ANTI-CANCER AGENTS
#1880METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS
#1881Nucleic acids for inhibiting expression of TMPRSS6 and iron chelators
#1882NOVEL EUKARYOTIC CELLS AND METHODS FOR RECOMBINANTLY EXPRESSING A PRODUCT OF INTEREST
#1883SMALL INTERFERING RNA (siRNA) FOR INHIBITING THE EXPRESSION OF MINI-CHROMOSOME MAINTENANCE 7 (MCM7) GENE, AND COMPOSITION AND USE THEREOF
#1884NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#1885T CELL RECEPTORS AND METHODS OF USE THEREOF
#1886Treatment Of Increased Lipid Levels With Sterol Regulatory Element Binding Protein Cleavage-Activating Protein (SCAP) Inhibitors
#1887Pharmaceutical composition for treatment and prevention of chronic disease
#1888BIO-PRODUCTION OF LENTIVIRAL VECTORS
#1889IMMUNE CELLS EXPRESSING RECEPTOR SPECIFIC TO CLASS I MHC MOLECULE AND INTERFERING RNA FOR BETA2 MICROGLOBULIN GENE
#1890NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND CONJUGATE, PREPARATION METHOD THEREFOR AND USE THEREOF
#1891Extended dicer substrate agents and methods for the specific inhibition of gene expression
#1892LNCRNAS FOR THERAPY AND DIAGNOSIS OF CARDIAC HYPERTROPHY
#1893Methods and Compositions for Selecting siRNA of Improved Functionality
#1894Gene-regulating compositions and methods for improved immunotherapy
#1895CD52-DEFICIENT CELLS FOR ADOPTIVE CELL THERAPY
#1896A PHARMACEUTICAL COMPOSITION OF S1PR MODULATORS
#1897Using fatty acid synthase inhibitors to treat fibrosis
#1898PLANT VIRAL NUCLEIC ACID DELIVERY PARTICLES AND USES THEREOF
#1899RECONSTRUCTING HUMAN EARLY EMBRYOGENESIS IN VITRO WITH PLURIPOTENT STEM CELLS
#1900ASSAYS AND METHODS FOR DETERMINING ACTIVITY OF A THERAPEUTIC AGENT IN A SUBJECT
#1901COMPOSITION FOR PREVENTING OR TREATING CANCER
#1902Treatment of liver disease with mitochondrial glycerol-3-phosphate acyltransferase (GPAM) inhibitors
#1903USES OF SYNTHETIC LETHAL PARTNERS FOR TREATMENT OF CANCER
#1904PROCESS OF DELIVERING SMALL RNAS TO SPERM
#1905DELIVERY OF OLIGONUCLEOTIDES TO THE STRIATUM
#1906RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF
#1907PROCESS FOR FORMULATING AN ANIONIC AGENT
#1908COMBINATION OF HEPATITIS B VIRUS (HBV) VACCINES AND HBV-TARGETING RNAI
#1909COMBINATION OF HEPATITIS B VIRUS (HBV) VACCINES AND HBV-TARGETING RNAi
#1910SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#1911METHODS OF TREATING CANCER WITH AN INHIBITOR OF ZNF827
#1912METHODS AND COMPOSITIONS FOR MICROBIAL DELIVERY OF DOUBLE STRANDED RNA
#1913SIRNA SEQUENCES TARGETING THE EXPRESSION OF HUMAN GENES JAK1 OR JAK3 FOR A THERAPEUTIC USE
#1914APPLICATION OF COMBINED INHIBITION OF LNCRNA SAMMSON AND BRAF KINASE IN DELAYING ADAPTIVE DRUG-RESISTANCE OF MELANOMA
#1915GALNAC CLUSTER PHOSPHORAMIDITE AND TARGETED THERAPEUTIC NUCLEOSIDES
#1916NOVEL EUKARYOTIC CELLS AND METHODS FOR RECOMBINANTLY EXPRESSING A PRODUCT OF INTEREST
#1917METHODS OF TREATING CANCERS CONTAINING FUSION GENES
#1918NUCLEIC ACID-CONTAINING LIPID PARTICLES AND RELATED METHODS
#1919Suppression of pathological angiogenesis by inhibition of NR2F6
#1920COMPOSITIONS AND METHODS FOR INHIBITING PCSK9
#1921A Method Of Promoting Survival And/Or Function Of A Motor Neuron And Related Agents, Uses And Methods
#1922Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#1923COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#1924USE OF MÜLLERIAN INHIBITING SUBSTANCE INHIBITORS FOR TREATING CANCER
#1925Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro
#1926Defined multi-conjugates oligonucleotides
#1927Modified RNA agents with reduced off-target effect
#1928Nucleic acids for inhibiting expression of LPA in a cell
#1929Products and compositions
#1930COMPOUNDS AND METHODS FOR REDUCING SPDEF EXPRESSION
#1931Muscle targeting complexes and uses thereof for treating dystrophinopathies
#1932CONJUGATES AND METHODS FOR TREATING ACROMEGALY
#1933GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#19342'-METHOXY SUBSTITUTED OLIGOMERIC COMPOUNDS AND COMPOSITIONS FOR USE IN GENE MODULATIONS
#1935High performance multi-input microRNA sensors and uses thereof
#1936CO-DELIVERY OF TGF-B siRNA AND PDL1 siRNA TO TREAT CANCER
#1937METHODS OF INDUCING INSULIN PRODUCTION
#1938Treatment of liver diseases with cell death inducing DFFA like effector B (CIDEB) inhibitors
#1939LONG NON-CODING RNA IN CANCER
#1940VH4 antibodies and compositions comprising the same
#1941METHODS OF TREATING P53 MUTANT CANCERS USING OGDH INHIBITORS
#1942METHOD AND COMPOSITION FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#1943Methods And Compositions For Enhancing AAV-Mediated Homologous Recombination Using Ribonucleotide Reductase Inhibitors
#1944Methods and compositions for targeting RNA polymerases and non-coding RNA biogenesis to specific loci
#1945TARGETING SLC38A2 IN PANCREATIC CANCER
#1946COMPOSITIONS AND METHODS FOR THE TREATMENT OF HYPERCHOLESTEROLEMIA
#1947Oligonucleotide interference treatments of prostate cancer
#1948METHODS AND COMPOSITIONS FOR TREATING MALIGNANT TUMORS ASSOCIATED WITH KRAS MUTATION
#1949USE OF RAB7 GTPASE (RAB7) INHIBITORS IN ENHANCING PERMEABILITY OF THE BLOOD BRAIN BARRIER (BBB)
#1950Striatin interacting protein inhibitor and use thereof in preparation of anti-tumor drug
#1951COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#1952RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING CHEMICALLY MODIFIED SHORT INTERFERING NUCLEIC ACID (SINA)
#1953T CELL RECEPTORS AND METHODS OF USE THEREOF
#1954Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1955Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1956Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1957COMPOSITIONS AND METHODS TO CONTROL INSECT PESTS
#1958CONJUGATES OF BILE ACIDS AND THEIR DERIVATIVES FOR ACTIVE MOLECULES DELIVERY
#1959SiRNA structures for high activity and reduced off target
#1960NUCLEIC ACID DRUG TARGETING MURF1
#1961METHODS FOR TREATING RAN PROTEIN-ASSOCIATED NEUROLOGICAL DISEASES
#1962CANCER TREATMENT USING TARGETED siRNA PHARMACEUTICAL FORMULATIONS TO DOWNREGULATE EXPRESSION OF PRDM14 PROTEIN
#1963COMPOSITIONS AND METHODS OF USING C/EBP ALPHA SARNA
#1964MEDICAL USES, METHODS AND USES
#1965METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#1966HSD17B13 variants and uses thereof
#1967Gene-regulating compositions and methods for improved immunotherapy
#1968BIODEGRADABLE CATIONIC POLYMERS AND USES THEREOF
#1969SPLICE MODULATING OLIGONUCLEOTIDES TARGETING RECEPTOR FOR ADVANCED GLYCATION END PRODUCTS AND METHODS OF USE
#1970COMPOSITIONS AND METHODS FOR THE TREATMENT OF LEUKODYSTROPHY AND WHOLE ANIMAL AND CELLULAR MODELS FOR IDENTIFYING EFFICACIOUS AGENTS FOR TREATMENT OF THE SAME
#1971Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1972INCREASING ATOH1 LIFE TO DRIVE SENSORINEURAL HAIR CELL DIFFERENTIANTION
#1973COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#1974OLIGONUCLEOTIDE ANTAGONISTS FOR RNA GUIDED GENOME EDITING
#1975CONTROL OF MAMMALIAN GENE DOSAGE USING CRISPR
#1976Anti-inflammatory treatment via inhibition of endothelial cell kinesin light chain 1, variant 1 (KLC1C)
#1977ANTI-INFECTION EFFECTS OF HNRNPA2B1 AND USE THEREOF
#1978Methods of Treating Transthyretin (TTR) Mediated Amyloidosis
#1979MUTANT CALRETICULIN FOR THE DIAGNOSIS OF MYELOID MALIGNANCIES
#1980COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#1981TREATMENT AND PREVENTION OF DISEASE MEDIATED BY WWP2
#1982Methods and compositions related to RNA-targeted Rho small GTPase RND3/RhoE therapy
#1983CELLS ENGINEERED FOR OLIGONUCLEOTIDE DELIVERY, AND METHODS FOR MAKING AND USING THEREOF
#1984Compositions and Methods for Reducing Perineural Invasion and Pain
#1985p16INK4a INHIBITOR FOR PREVENTING OR TREATING HUNTINGTON'S DISEASE
#1986EPH2A APTAMER AND USES THEREOF
#1987O-methyl rich fully stabilized oligonucleotides
#1988OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA
#1989PEGylated synthetic KL4 peptide, Compositions and Methods Thereof
#1990TRANSFECTION METHOD
#1991IMMUNOTHERAPEUTIC CONSTRUCTS AND METHODS OF THEIR USE
#1992SEX-LINKED RNAI INSECTICIDE MATERIALS AND METHODS
#1993Adeno-Associated Virus Virions with Variant Capsid and Methods of Use Thereof
#1994Compositions and Methods for Monitoring, Diagnosis, Detection and Treatment of Cancer
#1995NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#1996Lipid formulated compositions and methods for inhibiting expression of serum amyloid a gene
#1997COMPOSITIONS AND METHODS FOR PROVIDING CHEMOPROTECTIVE EFFECTS
#1998Conjugation of lipophilic albumin-binding moiety to RNA for improved carrier-free in vivo pharmacokinetics and gene silencing
#1999Compositions and methods for monitoring, diagnosis, prognosis, detection, and treatment of cancer
#2000RNAi Inhibition of Alpha-ENaC Expression
#2001NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#2002Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#2003GALANIN- AND GALANIN RECEPTOR BASED COMPOUNDS FOR THE TREATMENT OF LIVER FIBROSIS
#2004USE OF CD9 AS A BIOMARKER AND AS A BIOTARGET IN GLOMERULONEPHRITIS OR GLOMERULOSCLEROSIS
#2005Carboxypeptidase B2 (CPB2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2006Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA
#2007SERPIN FAMILY F MEMBER 2 (SERPINF2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2008OLIGONUCLEOTIDES FOR DGAT2 MODULATION
#2009COMPOUND, METHOD AND PHARMACEUTICAL COMPOSITION FOR MODULATING EXPRESSION OF DUX4
#2010NUCLEIC ACID MOLECULES ENCODING AN ENGINEERED ANTIGEN RECEPTOR AND AN INHIBITORY NUCLEIC ACID MOLECULE AND METHODS OF USE THEREOF
#2011THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#2012Compositions and methods for the delivery of nucleic acids
#2013METHODS AND COMPOSITIONS FOR MODULATION OF AN INTERSPECIES GUT BACTERIAL PATHWAY FOR LEVODOPA METABOLISM
#2014METHODS AND COMPOSITIONS FOR TREATING MELANOMA
#2015METHOD FOR INHIBITING INFECTION AND ACTIVATION OF VIRUS
#2016MODULATORS OF TELOMERE DISEASE
#2017METHODS OF TREATING DISEASES ASSOCIATED WITH CELLS EXHIBITING ER STRESS OR WITH NEURAL TISSUE DAMAGE
#2018MEDIATORS OF GENE SILENCING
#2019Treatment of liver diseases with cell death inducing DFFA like effector B (CIDEB) inhibitors
#2020Gene-regulating compositions and methods for improved immunotherapy
#2021METHOD OF PRODUCING MICROBIAL OIL CONTAINING FATTY ACIDS OBTAINED FROM STRAMENOPILE
#2022Method of treating aging-associated cognitive impairment by reducing CCR3
#2023COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2024TARGETING MISSPLICED TRANSCRIPTS IN GENETIC DISORDERS
#2025DUAL TARGETING siRNA AGENTS
#2026COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#2027Bruton's Tyrosine Kinase as Anti-Cancer Drug Target
#2028Treatment of amyotrophic lateral sclerosis (ALS)
#2029ORAL DELIVERY OF OLIGONUCLEOTIDES
#2030Nanoparticle to target cancer
#2031RNAi agents for inhibiting expression of HIF-2 alpha (), compositions thereof, and methods of use
#2032COMPOSITIONS AND METHODS FOR RAPID AND DYNAMIC FLUX CONTROL USING SYNTHETIC METABOLIC VALVES
#2033Genetically-modified immune cells comprising a microRNA-adapted shRNA (shRNAmiR)
#2034Agent for use in the treatment of glioma
#2035HIGH DENSITY LIPOPROTEIN BINDING PROTEIN (HDLBP/VIGILIN) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#2036RETROVIRAL VECTOR HAVING IMMUNE-STIMULATING ACTIVITY
#2037TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#2038NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL
#2039RNA interference mediated inhibition of gene expression using short interfering nucleic acids (siNA)
#2040COMPOSITIONS AND METHODS FOR TREATING RAS-MUTANT CANCERS
#2041Haploid induction compositions and methods for use therefor
#2042IMPROVEMENTS RELATING TO CELL TRANSFECTION
#2043ARGONAUTE PROTEINS FROM PROKARYOTES AND APPLICATIONS THEREOF
#2044METHODS AND COMPOSITIONS FOR INHIBITING EXPRESSION OF CYP27A1
#2045Therapeutic Targets for Oncogenic KRAS-Dependent Cancers
#2046CELL-PENETRATING PEPTIDES
#2047INHIBITION OF HISTONE METHYL TRANSFERASES TO TREAT CANCER
#2048Treatment and diagnosis of inflammatory disorders
#2049HIPK INHIBITORS AND METHODS OF USE THEREOF
#2050Modified short interfering nucleic acid (siNA) molecules and uses thereof
#2051ENDOSOMAL CLEAVABLE LINKERS
#2052Antisense Oligonucleotides Targeting ATXN3
#2053ENGINEERED EXOSOMES FOR TARGETED DELIVERY
#2054DOUBLE-STRANDED NUCLEIC ACID INHIBITOR MOLECULES WITH SHORTENED SENSE STRANDS
#2055HAIRPIN-LIKE OLIGONUCLEOTIDE-CONJUGATED SPHERICAL NUCLEIC ACID
#2056AIM2 INHIBITORS AND USES THEREOF
#2057Method for diagnosis of Alzheimer's disease using microrna
#2058COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
#2059RNAI MOLECULE
#2060CONTROL OF INSECT PESTS USING RNA MOLECULES
#2061IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#2062Nucleic acids for inhibiting expression of LPA in a cell
#2063Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use
#2064T CELL RECEPTORS AND METHODS OF USE THEREOF
#2065T CELL RECEPTORS AND METHODS OF USE THEREOF
#2066TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS AND DISORDERS ASSOCIATED WITH THE SPINAL CORD
#2067RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS
#2068Modulatory polynucleotides
#2069Extended dicer substrate agents and methods for the specific inhibition of gene expression
#2070COMPOSITIONS COMPRISING ALTERNATING 2'-MODIFIED NUCLEOSIDES FOR USE IN GENE MODULATION
#2071POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF
#2072OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#2073Mammalian somatic cell with modified RNA encoding reprogramming factors
#2074BIFUNCTIONAL VECTORS ALLOWING BCL11A SILENCING AND EXPRESSION OF AN ANTI-SICKLING HBB AND USES THEREOF FOR GENE THERAPY OF B-HEMOGLOBINOPATHIES
#2075SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
#2076Methods to identify and treat subjects having corticosteroid-resistant inflammatory diseases
#2077PROCESS CONTROL IN CELL BASED ASSAYS
#2078COMPOSITIONS AND METHODS FOR THE TREATMENT OF KRAS ASSOCIATED DISEASES OR DISORDERS
#2079NOVEL NUCLEIC ACID MOLECULES AND THEIR USE IN THERAPY
#2080CHMP2A as a Regulator of Natural Killer Cell-Mediated Activity
#2081T CELL RECEPTORS AND METHODS OF USE THEREOF
#2082Therapeutic targets for facioscapulohumeral muscular dystrophy
#2083RSK INHIBITORS IN THE TREATMENT OF VIRUS DISEASES
#2084FRAGILE X MENTAL RETARDATION PROTEIN INTERFERING OLIGONUCLEOTIDES AND METHODS OF USING SAME
#2085siRNA/Nanoparticle Formulations for Treatment of Middle-East Respiratory Syndrome Coronaviral Infection
#2086CTLA-4 aptamer conjugates
#2087Methods and compositions for increased double stranded RNA production
#2088Muscle targeting complexes and uses thereof for treating dystrophinopathies
#2089siRNA Inhibition Of Human Antigen R Expression For Treatment of Cancer
#2090TARGETED SENSITIZATION OF NON-DEL(5q) MALIGNANT CELLS
#2091Compositions for treating heart disease by inhibiting the action of mAKAP-β
#2092PREVENTION OR TREATMENT OF FIBROTIC DISEASE
#2093TARGETING SENESCENT CELLS
#2094DIAGNOSIS AND TREATMENT OF MEDULLOBLASTOMA
#2095NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#2096CORE MASTER REGULATORS OF GLIOBLASTOMA STEM CELLS
#2097NOVEL USE OF REGULATORY T CELL-SPECIFIC SURFACE PROTEIN LRIG-1
#2098Compositions and methods of treating muscle atrophy and myotonic dystrophy
#2099TARGETING MICRORNAS TO OVERCOME DRUG TOLERANCE AND RESISTANCE
#2100MODULATION OF CILIOGENESIS