109156 ⎘
Structure or type of the nucleic acid; Chemical structure of the backbone Phosphotriesters
IMMUNOMODULATING POLYNUCLEOTIDES, ANTIBODY CONJUGATES THEREOF, AND METHODS OF THEIR USE
#2NUCLEASE-MEDIATED GENOME EDITING OF PRIMARY CELLS AND RELATED KITS
#3EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#4TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF GENE TRANSCRIPTS
#5TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#6ANTISENSE OLIGONUCLEOTIDE-BASED PROGRANULIN AUGMENTATION THERAPY IN NEURODEGENERATIVE DISEASES
#7Pharmaceutical compositions comprising gene-corrected primary cells
#8IMMUNOMODULATING POLYNUCLEOTIDES, ANTIBODY CONJUGATES THEREOF, AND METHODS OF THEIR USE
#9Nuclease-mediated genome editing of primary cells
#10Antisense oligonucleotide-based progranulin augmentation therapy in neurodegenerative diseases
#11LNA-G process
#12TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#13Exosomal loading using hydrophobically modified oligonucleotides
#14Modulating RNA Interactions with Polycomb Repressive Complex 1 (PRC1)
#15Methods of selecting therapeutic molecules
#16POLYNUCLEOTIDE CONSTRUCTS HAVING AN AUXILIARY MOIETY NON-BIOREVERSIBLY LINKED TO AN INTERNUCLEOSIDE PHOSPHATE OR PHOSPHOROTHIOATE
#17LNA-G Process
#18TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#19Nuclease-mediated genome editing of primary cells and enrichment thereof
#20Immunomodulating polynucleotides, antibody conjugates thereof, and methods of their use
#21METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF MYC BY DOUBLE-STRANDED RNA
#22TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#23Exosomal loading using hydrophobically modified oligonucleotides
#24METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF MYC BY DOUBLE-STRANDED RNA
#25POLYNUCLEOTIDE CONSTRUCTS HAVING DISULFIDE GROUPS
#26Phosphorous-linked oligomeric compounds and their use in gene modulation
#27Modified cytosine polynucleotide oligomers and methods
#28Treatment of hepatocyte growth factor (HGF) related diseases by inhibition of natural antisense transcript to HGF
#29Neutral nucleic acid ligands
#30TREATMENT OF HEPATOCYTE GROWTH FACTOR (HGF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO HGF
#31Treatment of hepatocyte growth factor (HGF) related diseases by inhibition of natural antisense transcript to HGF
#32NUCLEIC ACID DELIVERY COMPOSITIONS AND METHODS OF USE THEREOF
#33TREATMENT OF GLIAL CELL DERIVED NEUROTROPHIC FACTOR (GDNF) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO GDNF
#34NOVEL SIRNA STRUCTURES
#35Phosphate-modified oligonucleotide analogs with enhanced immunostimulatory activity
#36OLIGORIBONUCLEOTIDES AND RIBONUCLEASES FOR CLEAVING RNA
#37HUMAN RNASE III AND COMPOSITIONS AND USES THEREOF
#38Interfering RNA duplex having blunt-ends and 3′-modifications
#39Antisense oligonucleotide to inhibit melanoma inhibitory activity, MIA
#40Inhibition of chronic myelogenous leukemic cell growth by liposomal-antisense oligodeoxy-nucleotides targeting to Grb2 or Crk1
#41Interfering Rna Duplex Having Blunt-Ends And 3'-Modifications
#42Three component chimeric antisense oligonucleotides
#43Human RNase III and compositions and uses thereof