ClassID:

109155

C12N2310/31 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Chemical structure of the backbone

Sub-classes:
Recent Application in this class:
#1
20260109986
2026-04-23

THERAPEUTIC OLIGONUCLEOTIDES TO CORRECT CYSTIC FIBROSIS MUTATIONS

#2
20260076989
2026-03-19

OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF

#3
20260035703
2026-02-05

Compositions and Methods for Correcting Limb Girdle Muscular Dystrophy Type 2C Using Exon Skipping

#4
20260035695
2026-02-05

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION

#5
20260021195
2026-01-22

RNAI AGENTS FOR INHIBITING EXPRESSION OF HUNTINGTIN (HTT), COMPOSITIONS THEREOF, AND METHODS OF USE

#6
20260015613
2026-01-15

FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#7
20260009035
2026-01-08

GALNAC COMPOUND CONTAINING RIBOSE RING OR ITS DERIVATIVE STRUCTURE AND OLIGONUCLEOTIDE CONJUGATE THEREOF

#8
20260002154
2026-01-01

COMPOUNDS AND METHODS FOR REDUCING PRION EXPRESSION

#9
20250381284
2025-12-18

PRNP RNAi AGENTS

#10
20250368992
2025-12-04

NUCLEIC ACID COMPOUNDS

#11
20250346899
2025-11-13

CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE

#12
20250340880
2025-11-06

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#13
20250333741
2025-10-30

Conjugated Antisense Compounds and Their Use

#14
20250333736
2025-10-30

BBB-CROSSING LIPID LIGAND OF HETERO NUCLEIC ACID

#15
20250313836
2025-10-09

CHIRAL DESIGN

#16
20250304613
2025-10-02

AMINOOXY CLICK CHEMISTRY (AOCC): A VERSATILE CONJUGATION APPROACH

#17
20250283085
2025-09-11

Oligonucleotide Terminal Phosphate Derivatives and Method of Use

#18
20250263704
2025-08-21

NUCLEIC ACID-POLYPEPTIDE NANO-PHARMACEUTICAL COMPOSTION FOR TREATING AND PREVENTING HUMAN PAPILLOMA VIRUS INFECTION

#19
20250263693
2025-08-21

Guide RNA Constructs for Therapeutic Gene Editing

#20
20250255897
2025-08-14

P-ETHOXY NUCLEIC ACIDS FOR LIPOSOMAL FORMULATION

#21
20250243492
2025-07-31

COMPOSITIONS AND METHODS FOR TREATMENT OF PRION DISEASES

#22
20250207128
2025-06-26

POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF

#23
20250205272
2025-06-26

MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT

#24
20250197864
2025-06-19

LNCRNA TRANSCRIPTS IN MELANOMAGENESIS

#25
20250188470
2025-06-12

MULTIPLEXING TARGETING LIGANDS THROUGH CLICK CHEMISTRY AT THE ANOMERIC SITE OF SUGARS

#26
20250188463
2025-06-12

ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF

#27
20250179491
2025-06-05

ATXN2 RNA INTERFERENCE AGENTS

#28
20250146024
2025-05-08

Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription

#29
20250122537
2025-04-17

Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription

#30
20250115907
2025-04-10

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA

#31
20250092404
2025-03-20

PIKFYVE ANTISENSE OLIGONUCLEOTIDES

#32
20250051776
2025-02-13

COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS ASSOCIATED WITH ARDS INDUCED PULMONARY FIBROSIS

#33
20250051766
2025-02-13

TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE TRANSCRIPTS

#34
20240425852
2024-12-26

Pan-Genotypic Agents Against Influenza Virus and Methods of Using the Same

#35
20240417756
2024-12-19

Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription

#36
20240401038
2024-12-05

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION

#37
20240360452
2024-10-31

METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50-53

#38
20240352455
2024-10-24

Compositions and methods for modulating apolipoprotein (a) expression

#39
20240309382
2024-09-19

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#40
20240301428
2024-09-12

COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING

#41
20240301422
2024-09-12

COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION

#42
20240294923
2024-09-05

Selective Antisense Compounds and Uses Thereof

#43
20240287522
2024-08-29

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#44
20240279664
2024-08-22

Conjugated antisense compounds and their use

#45
20240247260
2024-07-25

CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE

#46
20240229026
2024-07-11

CHIRAL CONTROL

#47
20240218363
2024-07-04

OPTIMIZED 2'- MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE

#48
20240200076
2024-06-20

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#49
20240182892
2024-06-06

DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS

#50
20240091383
2024-03-21

SYNERGISTIC EFFECT OF SMN1 AND MIR-23A IN TREATING SPINAL MUSCULAR ATROPHY

#51
20240076664
2024-03-07

FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#52
20240018515
2024-01-18

COMPLEMENT FACTOR B (CFB) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#53
20230407305
2023-12-21

Oligonucleotides conjugated to oleic acid and uses thereof

#54
20230374519
2023-11-23

COMPOUNDS AND METHODS FOR MODULATING PMP22

#55
20230340475
2023-10-26

OLIGONUCLEOTIDES FOR MLH1 MODULATION

#56
20230340474
2023-10-26

Compositions and methods of treating facioscapulohumeral muscular dystrophy

#57
20230295622
2023-09-21

COMPOSITIONS AND METHODS FOR SILENCING MYOC EXPRESSION

#58
20230287420
2023-09-14

Compositions and methods of treating facioscapulohumeral muscular dystrophy

#59
20230279395
2023-09-07

Compositions and methods of treating Facioscapulohumeral muscular dystrophy

#60
20230272401
2023-08-31

COMPOSITIONS FOR FLCN GENE MODULATION AND METHODS THEREOF

#61
20230256001
2023-08-17

MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT

#62
20230242918
2023-08-03

INTERFERON- INDUCING OLIGONUCLEOTIDE DUPLEXES AND METHODS OF USE

#63
20230227826
2023-07-20

UNA OLIGOMERS FOR THE TREATMENT OF POLYGLUTAMINE DISEASES

#64
20230220390
2023-07-13

NUCLEIC ACID MOLECULE HAVING IMPROVED STABILITY, AND USE THEREOF

#65
20230212614
2023-07-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA DIRECTED MODULATION OF TRANSCRIPTION

#66
20230212583
2023-07-06

ANTISENSE THERAPEUTICS FOR THE TREATMENT OF CORONAVIRUS

#67
20230167452
2023-06-01

COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING

#68
20230159923
2023-05-25

RIG-I Agonists and Methods of Using Same

#69
20230151365
2023-05-18

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#70
20230147979
2023-05-11

DESIGN METHOD FOR OPTIMIZED RIG-I LIGANDS

#71
20230129651
2023-04-27

HAIRPIN STRUCTURE NUCLEIC ACID MOLECULES CAPABLE OF MODULATING TARGET GENE EXPRESSION AND USES THEREOF

#72
20230108357
2023-04-06

Polymerizable compound, compound, and method for producing boranophosphate oligomer

#73
20230104708
2023-04-06

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#74
20230095566
2023-03-30

ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS

#75
20230064031
2023-03-02

4′-phosphate analogs and oligonucleotides comprising the same

#76
20230032974
2023-02-02

SMALL RIBOSOMAL PROTEIN SUBUNIT 25 (RPS25) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#77
20230002771
2023-01-05

Compounds and methods for modulating factor XII

#78
20220411804
2022-12-29

PIKFYVE antisense oligonucleotides

#79
20220401467
2022-12-22

OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF

#80
20220315923
2022-10-06

COMPOUNDS AND METHODS FOR REDUCING SNCA EXPRESSION

#81
20220307019
2022-09-29

DOUBLE-STRANDED NUCLEIC ACID COMPLEX AND USE THEREOF

#82
20220290150
2022-09-15

Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro

#83
20220290141
2022-09-15

ANTISENSE OLIGONUCLEOTIDE THERAPY FOR CANCER

#84
20220275365
2022-09-01

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#85
20220267928
2022-08-25

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#86
20220267808
2022-08-25

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#87
20220267807
2022-08-25

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#88
20220259620
2022-08-18

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#89
20220259592
2022-08-18

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#90
20220243200
2022-08-04

COMPOSITIONS AND METHODS FOR MODULATING TAU EXPRESSION

#91
20220243198
2022-08-04

Pan-Genotypic Agents Against Influenza Virus and Methods of Using the Same

#92
20220228140
2022-07-21

COMPOUND, METHOD AND PHARMACEUTICAL COMPOSITION FOR MODULATING EXPRESSION OF DUX4

#93
20220162602
2022-05-26

POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF

#94
20220127608
2022-04-28

P-ethoxy nucleic acids for STAT3 inhibition

#95
20220119820
2022-04-21

COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING

#96
20220119439
2022-04-21

5'-Cyclo-Phosphonate Modified Nucleotides

#97
20220112521
2022-04-14

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

#98
20220049276
2022-02-17

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#99
20220042013
2022-02-10

Compositions and their uses directed to huntingtin

#100
20220033817
2022-02-03

Targeting Ligands

#101
20220025407
2022-01-27

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#102
20220025366
2022-01-27

Compounds and methods for reducing prion expression

#103
20220010338
2022-01-13

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#104
20220002724
2022-01-06

AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#105
20210395734
2021-12-23

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION

#106
20210388395
2021-12-16

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#107
20210388394
2021-12-16

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#108
20210369762
2021-12-02

Compositions and methods of treating Facioscapulohumeral muscular dystrophy

#109
20210361695
2021-11-25

P-ethoxy nucleic acids for liposomal formulation

#110
20210340575
2021-11-04

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#111
20210332391
2021-10-28

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#112
20210332390
2021-10-28

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#113
20210301290
2021-09-30

Compositions and methods of treating Facioscapulohumeral muscular dystrophy

#114
20210269804
2021-09-02

MULTIPLEXED SHRNAS AND USES THEREOF

#115
20210261972
2021-08-26

Combination therapy with liposomal antisense oligonucleotides

#116
20210246447
2021-08-12

Factor XII (Hageman Factor) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), and Kininogen 1 (KNG1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#117
20210230639
2021-07-29

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#118
20210230600
2021-07-29

Nucleic acid-drug complex and use thereof

#119
20210230596
2021-07-29

RIG-I Agonists and Methods of Using Same

#120
20210228615
2021-07-29

Oligonucleotide compositions and methods thereof

#121
20210222205
2021-07-22

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#122
20210214725
2021-07-15

COMPOSITIONS FOR MODULATING EXPRESSION OF C9ORF72 ANTISENSE TRANSCRIPT

#123
20210163934
2021-06-03

BBB-crossing lipid ligand of hetero nucleic acid

#124
20210162011
2021-06-03

Methods for Improving Leptin Sensitivity for the Treatment of Obesity and Diabetes

#125
20210139911
2021-05-13

ANTISENSE COMPOSITION AND METHOD FOR TREATING MUSCLE ATROPHY

#126
20210130823
2021-05-06

COMPOSITIONS AND METHODS

#127
20210130821
2021-05-06

Chiral control

#128
20210123058
2021-04-29

P-ethoxy nucleic acids for BCL2 inhibition

#129
20210115451
2021-04-22

P-ETHOXY NUCLEIC ACIDS FOR IGF-1R INHIBITION

#130
20210115444
2021-04-22

Chiral design

#131
20210108231
2021-04-15

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#132
20210102201
2021-04-08

Method of nonspecific target capture of nucleic acids

#133
20210095283
2021-04-01

HETERODUPLEX NUCLEIC ACID MOLECULES AND USES THEREOF

#134
20210087588
2021-03-25

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#135
20210087566
2021-03-25

Compositions and methods for modulating apolipoprotein (a) expression

#136
20210079428
2021-03-18

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#137
20210062226
2021-03-04

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#138
20210062225
2021-03-04

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#139
20210062224
2021-03-04

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#140
20210062223
2021-03-04

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#141
20210032631
2021-02-04

Compositions and Methods for Correcting Limb Girdle Muscular Dystrophy Type 2C Using Exon Skipping

#142
20210024923
2021-01-28

COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION

#143
20210024915
2021-01-28

METHOD FOR ACTIVATING P21 GENE EXPRESSION

#144
20210017522
2021-01-21

COMPOSITIONS AND THEIR USES DIRECTED TO HUNTINGTIN

#145
20200392509
2020-12-17

Conjugated antisense compounds and their use

#146
20200392498
2020-12-17

POLYNUCLEOTIDE CONSTRUCTS HAVING BIOREVERSIBLE AND NON-BIOREVERSIBLE GROUPS

#147
20200392494
2020-12-17

Compounds and methods for reducing SNCA expression

#148
20200385717
2020-12-10

Modulation of exon recognition in pre-mRNA by interfering with the secondary RNA structure

#149
20200362370
2020-11-19

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#150
20200362347
2020-11-19

Antisense oligonucleotides targeting alpha-synuclein and uses thereof

#151
20200362335
2020-11-19

Peptide phosphorodiamidate morpholino oligomers plant delivery to reduce pathogens and insect pests

#152
20200354749
2020-11-12

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#153
20200354748
2020-11-12

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#154
20200354747
2020-11-12

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#155
20200339991
2020-10-29

Amyloid precursor protein (APP) RNAi agent compositions and methods of use thereof

#156
20200339985
2020-10-29

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

#157
20200325478
2020-10-15

Methods and compositions for modulating gene expression using oligonucleotide based drugs administered in vivo or in vitro

#158
20200318116
2020-10-08

Compositions and their uses directed to huntingtin

#159
20200299734
2020-09-24

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#160
20200299733
2020-09-24

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#161
20200263179
2020-08-20

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA

#162
20200263173
2020-08-20

Compositions and methods for treating transposon associated diseases

#163
20200248177
2020-08-06

SMALL GUIDE ANTISENSE NUCLEIC ACID AND USE THEREOF

#164
20200239886
2020-07-30

Methods and means for efficient skipping of exon 45 in Duchenne muscular dystrophy pre-mRNA

#165
20200239880
2020-07-30

Pan-genotypic agents against influenza virus and methods of using the same

#166
20200224198
2020-07-16

COMPOSITIONS AND METHODS FOR MODULATING HBV EXPRESSION

#167
20200199589
2020-06-25

Compounds and methods for reducing Tau expression

#168
20200190542
2020-06-18

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#169
20200131513
2020-04-30

Factor XII (hageman factor) (F12), kallikrein B, plasma (fletcher factor) 1 (KLKB1), and kininogen 1 (KNG1) iRNA compositions and methods of use thereof

#170
20200123546
2020-04-23

ANTISENSE NUCLEIC ACID FOR TREATING AMYOTROPHY

#171
20200113928
2020-04-16

P-ethoxy nucleic acids for liposomal formulation

#172
20200095583
2020-03-26

Methods and compositions for managing vascular conditions

#173
20200095578
2020-03-26

POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF

#174
20200080113
2020-03-12

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#175
20200056187
2020-02-20

SELECTIVE ANTISENSE COMPOUNDS AND USES THEREOF

#176
20200040339
2020-02-06

P-ethoxy nucleic acids for STAT3 inhibition

#177
20200032271
2020-01-30

Combination therapy with liposomal antisense oligonucleotides

#178
20200002703
2020-01-02

Aptamers for personal care applications

#179
20190383797
2019-12-19

Methods of selecting therapeutic molecules

#180
20190367914
2019-12-05

Conjugated antisense compounds and their use

#181
20190359979
2019-11-28

Oligomeric compounds comprising α-β-constrained nucleic acid

#182
20190330662
2019-10-31

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#183
20190323012
2019-10-24

TNF-alpha-binding aptamer, and therapeutic use for same

#184
20190323009
2019-10-24

Piston arrangement

#185
20190309295
2019-10-10

Treatment of collagen gene related diseases by inhibition of natural antisense transcript to a collagen gene

#186
20190309292
2019-10-10

Compounds and methods for enhanced cellular uptake

#187
20190284583
2019-09-19

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#188
20190271008
2019-09-05

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#189
20190270765
2019-09-05

Polymerizable compound, compound, and method for producing boranophosphate oligomer

#190
20190264236
2019-08-29

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#191
20190264235
2019-08-29

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#192
20190264234
2019-08-29

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#193
20190264233
2019-08-29

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#194
20190256871
2019-08-22

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#195
20190256870
2019-08-22

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#196
20190256869
2019-08-22

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#197
20190256849
2019-08-22

Targeting ligands

#198
20190249180
2019-08-15

Compositions and methods for correcting limb girdle muscular dystrophy type 2C using exon skipping

#199
20190225964
2019-07-25

MODULATION OF EXON RECOGNITION IN PRE-MRNA BY INTERFERING WITH THE SECONDARY RNA STRUCTURE

#200
20190209604
2019-07-11

Oligonucleotides, compositions and methods thereof

#201
20190177729
2019-06-13

4'-phosphate analogs and oligonucleotides comprising the same

#202
20190169649
2019-06-06

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#203
20190169648
2019-06-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

#204
20190169647
2019-06-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

#205
20190169646
2019-06-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

#206
20190169645
2019-06-06

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

#207
20190169644
2019-06-06

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#208
20190169643
2019-06-06

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#209
20190169642
2019-06-06

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

#210
20190169641
2019-06-06

Methods and compositions or RNA-directed target DNA modification and for RNA-directed modulation of transcription

#211
20190112602
2019-04-18

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