109193 ⎘
Structure or type of the nucleic acid; Chemical structure; Nature of the modification Conjugate
ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#302NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#303GALNAC-MONOMERS AND GALNAC-NUCLEIC ACID CONJUGATES
#304NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF
#305CONJUGATE OF SAPONIN, OLIGONUCLEOTIDE AND GALNAC
#306BLOCK COPOLYMERS
#307TOPICAL DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#308PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#309MODULATION OF PREKALLIKREIN (PKK) EXPRESSION
#310COMPOUNDS AND METHODS FOR INCREASING STMN2 EXPRESSION
#311TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#312COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE
#313SMALL INTERFERING RNA TARGETING HBV AND USES THEREOF
#314SMALL INTERFERING RNA TARGETING APOC3 AND USES THEREOF
#315DOUBLE-STRANDED OLIGONUCLEOTIDE, COMPOSITION AND CONJUGATE CONTAINING DOUBLE-STRANDED OLIGONUCLEOTIDE, AND PREPARATION METHODS AND USES
#316COMPOSITIONS AND METHODS FOR TREATING OR PREVENTING STARGARDT'S DISEASE AND/OR RETINAL BINDING PROTEIN 4 (RBP4)-ASSOCIATED DISORDERS
#317METABOLIC DISORDER-ASSOCIATED TARGET GENE IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#318COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING
#319METHODS AND COMPOSITIONS FOR TREATING CHRONIC LIVER DISEASE AND HEPATOCELLULAR CARCINOMA
#320COMPOUNDS FOR MODULATING UNC13A EXPRESSION
#321OLIGONUCLEOTIDES FOR HTT-1A MODULATION
#322COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)
#323Selective Antisense Compounds and Uses Thereof
#324SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#325Oligonucleotides for Modulating Apolipoprotein E4 Expression
#326COMPLEMENT COMPONENT C3 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#327SELECTIVE DELIVERY OF OLIGONUCLEOTIDES TO GLIAL CELLS
#328CARBOHYDRATE CONJUGATES FOR THE DELIVERY OF THERAPEUTIC OLIGONUCLEOTIDES
#329COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM
#330GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#331TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#332METHOD FOR SYNTHESIS OF LINKAGE MODIFIED OLIGOMERIC COMPOUNDS
#333TREATMENT OF MTRES1 RELATED DISEASES AND DISORDERS
#334RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#335COMPOSITIONS AND METHODS OF TREATING DISEASES ASSOCIATED WITH BILE ACID TRANSPORTER
#336METHODS OF TREATING ALZHEIMER'S DISEASE
#337Conjugated antisense compounds and their use
#338TREATMENT OF ANGPTL4 RELATED DISEASES
#339DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#340LIGAND-BINDING NUCLEIC ACID COMPLEX
#341FOLLICULIN iRNA COMPOSITIONS AND METHODS THEREOF
#342RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#343SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#344POLYNUCLEIC ACID MOLECULES TARGETING PCSK9 AND USES THEREOF
#345COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF HEPATITIS B VIRUS (HBV)PROTEIN
#346LPA INHIBITOR AND USE THEREOF
#347COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#348COMPOSITION COMPRISING AN RNA THERAPEUTIC TARGETING FAT10 AND USES OF SAME FOR TREATING DISORDERS CHARACTERIZED BY ABNORMAL LIPID ACCUMULATION
#349Methods and Compositions for Adar-Mediated Editing
#350MODULATION OF COASY EXPRESSION
#351Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#352COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#353SIRNAS TARGETING SLC10A1 TRANSCRIPTS, COMPOSITIONS AND USES THEREOF
#354METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#355CARBOHYDRATE CONJUGATED RNA AGENTS AND PROCESS FOR THEIR PREPARATION
#356METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#357CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#358TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#359SIRNA TARGETING TMPRSS6 FOR THE TREATMENT OF MYELOPROLIFERATIVE DISORDERS
#360APTAMER-TYPE MULTI-WARHEAD COVALENT DRUG
#361OPTIMIZED 2'- MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE
#362MODULATING APOLIPOPROTEIN (A) EXPRESSION
#363Aptamers For Personal Health Care Applications
#364PROLINE DEHYDROGENASE 2 (PRODH2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#365NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#366ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#367NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF A TARGET GENE COMPRISING PHOSPHORODITHIOATE LINKAGES
#368EXPANDING THE CHEMICAL SUBSTRATES FOR GENETIC CODE REPROGRAMMING
#369DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES
#370ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#371RNA SILENCING AGENTS AND METHODS OF USE
#372NOVEL PEPTIDE-OLIGONUCLEOTIDE CONJUGATE AND USE THEREOF
#373USE OF MICRORNA-146A AND NANOCERIA CONJUGATE TO IMPROVE WOUND HEALING AND PROMOTE TISSUE REGENERATION
#374TRANSMEMBRANE PROTEASE, SERINE 6 (TMPRSS6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#375METHODS AND COMPOSITIONS FOR INHIBITING EXPRESSION OF LDHA
#376ENHANCED OLIGONUCLEOTIDES FOR INHIBITING RTELl EXPRESSION
#377TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#378METHODS FOR MODULATING FMR1 EXPRESSION
#379COMPOSITIONS OF MODIFIED TREMS AND USES THEREOF
#380Skeletal Muscle Delivery Platforms and Methods of Use
#381ANTISENSE OLIGONUCLEOTIDE
#382RNAi agents for inhibiting expression of complement component C3 (C3), pharmaceutical compositions thereof, and methods of use
#383CHEMICAL TOOLS FOR RNA 3D STRUCTURE DETERMINATION IN VIVO
#384Transcriptome In Vivo Analysis (TIVA) and Transcriptome In Situ Analysis (TISA)
#385KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#386KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#387SOLUTE CARRIER FAMILY MEMBER IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#388ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE
#389TARGETED INHIBITION USING ENGINEERED OLIGONUCLEOTIDES
#390Selective Antisense Compounds and Uses Thereof
#391ANTI-C5 AGENT FOR TREATMENT OF DRY AGE-RELATED MACULAR DEGENERATION (AMD) OR GEOGRAPHIC ATROPHY SECONDARY TO DRY AMD
#392Factor XII (F12) iRNA compositions and methods of use thereof
#393MODIFIED OLIGONUCLEOTIDES TARGETING SNPs
#394CATIONIC AMPHIPHILIC POLYMERS FOR CODELIVERY OF HYDROPHOBIC AGENTS AND NUCLEIC ACIDS
#395POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF
#396CONJUGATED OLIGONUCLEOTIDE COMPOUNDS, METHODS OF MAKING AND USES THEREOF
#397METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS
#398COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#399NOVEL LIGANDS FOR ASIALOGLYCOPROTEIN RECEPTOR
#400OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#401ANTISENSE OLIGOMERS TARGETING PCSK9
#402CONJUGATED OLIGONUCLEOTIDES
#403GENE CORRECTION OF POMPE DISEASE AND OTHER AUTOSOMAL RECESSIVE DISORDERS VIA RNA-GUIDED NUCLEASES
#404Compositions, systems, and methods for regulation of hepatitis B virus through targeted gene repression
#405Compositions, systems, and methods for regulation of hepatitis b virus through targeted gene repression
#406ORAL DELIVERY OF ANTISENSE CONJUGATES TARGETING PCSK9
#407NOVEL FATTY ACIDS AND THEIR USE IN CONJUGATION TO BIOMOLECULES
#408ANTISENSE COMPOUNDS
#409FN3 Domain-siRNA Conjugates with Enzyme Replacement Therapy
#410Oligomers and oligomer conjugates
#411RNA COMPOSITIONS AND METHODS FOR INHIBITING LIPOPROTEIN(A)
#412COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#413OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
#414GALNAC COMPOSITIONS FOR IMPROVING SIRNA BIOAVAILABILITY
#415Stabilized saRNA Compositions and Methods of Use
#416LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#417COMPLEX OF BETA-GLUCAN AND NUCLEIC ACID HAVING CONTROLLED PARTICLE SIZE
#418COMPOSITIONS AND METHODS FOR INHIBITING SNCA EXPRESSION
#419COMPOSITIONS AND METHODS FOR INHIBITING MAPT EXPRESSION
#420METHODS AND COMPOSITIONS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#421NUCLEIC ACIDS CONTAINING ABASIC NUCLEOTIDES
#422NOVEL EFFICACIOUS MICRORNA-30C ANALOGS REDUCE APOLIPOPROTEIN B SECRETION IN HUMAN LIVER CELLS
#423EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#424NUCLEIC ACID NANOSTRUCTURES FOR DELIVERY OF NUCLEIC ACID SEQUENCES TO CELLS
#425METHODS AND COMPOSITIONS FOR TREATING PRIMARY HYPEROXALURIA
#426MODIFIED GAPMER OLIGOMERS AND METHODS OF USE THEREOF
#427NOVEL RNA COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3
#428COMPOSITIONS AND METHODS FOR MODULATING SCAP ACTIVITY
#429COMPOUNDS AND METHODS FOR MODULATING PMP22
#430Effect of Fuel Doping in ICF Targets
#431Modified short interfering nucleic acid (siNA) molecules and uses thereof
#432SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#433Methods for treating or preventing ophthalmological conditions
#434METHODS FOR TREATING OR PREVENTING OPHTHALMOLOGICAL CONDITIONS
#435COMPOSITIONS AND METHODS FOR MODULATING COMPLEMENT FACTOR B EXPRESSION
#436Nucleic acid, composition and conjugate containing same, preparation method, and use thereof
#437ANTISENSE OLIGONUCLEOTIDES FOR MODULATION OF LONG NONCODING RNAS
#438SHORT INTERFERING NUCLEIC ACID (siNA) COMPOSITIONS
#439COMPOSITIONS AND METHODS FOR INHIBITING MITOCHONDRIA AMIDOXIME REDUCING COMPONENT 1 (MARC1) EXPRESSION
#440COMPOSITIONS AND METHODS FOR THE TREATMENT OF METABOLIC SYNDROME
#441ANAPLASTIC LYMPHOMA KINASE (ALK) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#442MAPT RNA interference agents
#443RNA-editing oligonucleotides and uses thereof
#444COMPOSITIONS COMPRISING LINEAR POLYRIBONUCLEOTIDES FOR PROTEIN MODULATION AND USES THEREOF
#445Amphiregulin gene-specific double-stranded oligonucleotide and composition for preventing and treating fibrosis-related diseases and respiratory diseases, comprising same
#446Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#447IRNA COMPOSITIONS AND METHODS FOR SILENCING GROWTH FACTOR RECEPTOR BOUND PROTEIN 10 (GRB10) OR GROWTH FACTOR RECEPTOR BOUND PROTEIN 14 (GRB14) IN THE LIVER
#448OLIGONUCLEOTIDES FOR REDUCTION OF PD-L1 EXPRESSION
#449Ketohexokinase (KHK) iRNA compositions and methods of use thereof
#450TUMOR NECROSIS FACTOR RECEPTOR ASSOCIATED FACTOR 6 (TRAF6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#451ANTIVIRAL SILENCING RNA MOLECULES, CHEMICALLY MODIFIED ANTIVIRAL SILENCING RNA MOLECULES WITH ENHANCED CELL PENETRATING ABILITIES, PHARMACEUTICAL COMPOSITIONS COMPRISING SAME AND USES THEREOF FOR TREATMENT OF VIRAL INFECTIONS
#452RNAi Agents And Compositions for Inhibiting Expression of Apolipoprotein C-III (APOC3)
#453Polynucleotides containing a morpholino linker
#454MONOCLONAL ANTIBODIES TO CHEMICALLY-MODIFIED NUCLEIC ACIDS AND USES THEREOF
#455MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR OVARIAN CANCER
#456POLYNUCLEOTIDE AGENTS TARGETING ANGIOTENSINOGEN (AGT) AND METHODS OF USE THEREOF
#457GROWTH AND SITE-SPECIFIC ORGANIZATION OF MICRO-SCALE BIMOLECULAR DEVICES ON LIVING CELLS
#458ANTI-SEED PNAS AND MICRORNA INHIBITION
#459Oligonucleotides for inducing paternal UBE3A expression
#460Targeted inhibition using engineered oligonucleotides
#461LIGAND COMPOUNDS, CONJUGATES, AND APPLICATIONS THEREOF
#462COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3 EXPRESSION
#463MAGNETIC INORGANIC IRON-BASED NANOPARTICLES
#464ANTI-C5 AGENT FOR TREATMENT OF DRY AGE-RELATED MACULAR DEGENERATION (AMD) OR GEOGRAPHIC ATROPHY SECONDARY TO DRY AMD
#465ORTHOGONALLY LINKED MULTIMERIC OLIGONUCLEOTIDES
#466Compositions and methods for modulating APOC3 expression
#467PRODUCTS AND COMPOSITIONS
#468Circular siRNAs
#469MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT
#470PCSK9 TARGETING OLIGONUCLEOTIDES FOR TREATING HYPERCHOLESTEROLEMIA AND RELATED CONDITIONS
#471COMPOUNDS AND METHODS FOR REDUCING MSH3 EXPRESSION
#472CONJUGATE OF DOUBLE-STRANDED SIRNA ANALOGUE
#473NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#474COMPOSITIONS AND METHODS FOR INHIBITING NUCLEAR RECEPTOR SUBFAMILY 1 GROUP H MEMBER 3 (NR1H3) EXPRESSION
#475Transmembrane protease, serine 6 (TMPRSS6) iRNA compositions and methods of use thereof
#476OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#477MAPT RNA INTERFERENCE AGENTS
#478SINGLE-STRANDED OLIGONUCLEOTIDE
#479AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#480DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#481CYTOTOXIC T-LYMPHOCYTE BINDING APTAMERS
#482BISPECIFIC PERSONALIZED APTAMERS
#483USE OF SBDS INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#484Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#485COMPOSITIONS FOR TRANSFER OF CARGO TO CELLS
#486Modified double-stranded RNA agents
#487COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING
#488COMPOUNDS AND METHODS FOR REDUCING PSD3 EXPRESSION
#489METHOD OF STIMULATING PROLIFERATION OF A CELL
#490COMPOSITIONS FOR TREATING CANCER WITH KRAS MUTATIONS AND USES THEREOF
#491MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#492Prekallikrein-modulating compositions and methods of use thereof
#493Selectively controllable cleavable linkers
#494COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#495NUCLEIC ACID COMPLEX AND PHARMACEUTICAL COMPOSITION CONTAINING SAME
#496OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#4971'-ALKYL MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE
#498Targeted Inhibition Using Engineered Oligonucleotides
#499MANNAN BINDING LECTIN SERINE PEPTIDASE 2 (MASP2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#500RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#501ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#502OLIGONUCLEOTIDES FOR MODULATING CD73 EXON 7 SPLICING
#503USE OF COPS3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#504COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#505MASKED FLUOROGENIC COMPOUNDS AND METHODS OF USING THE SAME
#506HYPERBRANCHED POLYMERS AND POLYPLEXES AND DNA OR RNA DELIVERY SYSTEMS INCLUDING THE SAME
#507COMPOSITIONS AND METHODS FOR MODULATING GROWTH HORMONE RECEPTOR EXPRESSION
#508USE OF SCAMP3 INHIBITORS FOR TREATING HEPATITIS B VIRUS INFECTION
#509NANOPARTICLES FOR EXPRESSION OF GENES OF INTEREST AND/OR REGULATION OF SIGNALING PATHWAYS
#510SYNTHETIC PROCESSES AND INTERMEDIATES
#511Selective Antisense Compounds and Uses Thereof
#512Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for treating hepatitis B infection
#513Transthyretin (TTR) iRNA compositions and methods of use thereof
#514METHOD FOR PREPARING MRNA-GALNAC TARGETING MOLECULE, IN VIVO DELIVERY SYSTEM THEREFOR, AND USE THEREOF
#515MODIFIED DOUBLE-STRANDED RNA AGENTS
#516COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-1 ANTITRYPSIN EXPRESSION
#517POLY(BETA-AMINO ESTER)-CO-POLYETHYLENE GLYCOL (PEG-PBAE-PEG) POLYMERS FOR GENE AND DRUG DELIVERY
#518PRODRUG INCORPORATED sgRNA SYNTHESIS
#519RNA-Editing Oligonucleotides and Uses Thereof
#520EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#521KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#522ANTI-ADAM33 OLIGONUCLEOTIDES AND RELATED METHODS
#523STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#524COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSING OF METHYLATION-CONTROLLED J-PROTEIN (MCJ)
#525ANTISENSE MOLECULES AND METHODS FOR TREATING PATHOLOGIES
#526Compositions and methods for modulating complement factor B expression
#527CTGF GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE, AND A COMPOSITION FOR PREVENTING AND TREATING FIBROTIC DISEASES AND RESPIRATORY-RELATED DISEASES COMPRISING SAME
#528Compositions and methods for inhibiting mitochondria amidoxime reducing component 1 (MARC1) expression
#529COMPOSITIONS AND METHODS FOR SILENCING DNAJB1-PRKACA FUSION GENE EXPRESSION
#530TARGETING GLIOBLASTOMA STEM CELLS THROUGH THE TLX-TET3 AXIS
#531APOLIPOPROTEIN B ANTAGONIST
#532COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#533Nucleic acids for inhibiting expression of C3 in a cell
#534NOVEL RNA THERAPEUTICS AND USES THEREOF
#535Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#536Oligonucleotides for SARS-CoV-2 modulation
#537Nucleic acids for inhibiting expression of PROS1 in a cell
#538RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#539RNAi Agents for Inhibiting Expression of Beta-ENaC, Compositions Thereof, and Methods of Use
#540METHODS FOR CONTROLLING EXTRACORPOREAL MEMBRANE OXYGENATION (ECMO) COAGULATION
#541RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#542COMBINATION THERAPY FOR C3 INHIBITION
#543PCSK9 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#544APTAMER NUCLEIC ACID MOLECULE, AND COMPLEX AND APPLICATION THEREOF
#545METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#546XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#547Twist signaling inhibitor compositions and methods of using the same
#548Modulation of Angiopoietin-Like 3 Expression
#549Oligonucleotide Progranulin Agonists
#550COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#551Trialkyne linking agents and methods of use
#552REFILLABLE DRUG DELIVERY DEVICES AND METHODS OF USE THEREOF
#553OLIGONUCLEOTIDES, COMPOSITIONS AND METHODS THEREOF
#554CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT
#555Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof
#556Modified double-stranded RNA agents
#557CONJUGATES AND METHODS FOR TREATING LIVER FIBROSIS
#558Xanthine dehydrogenase (XDH) iRNA compositions and methods of use thereof
#559DNA aptamers and use thereof for the treatment of cancer
#560Carbohydrate conjugate RNA agents and process for their preparation
#561Dynamic pharmacokinetic-modifying anchors
#562ANTI-C5 AGENT FOR TREATMENT OF DRY AGE-RELATED MACULAR DEGENERATION (AMD) OR GEOGRAPHIC ATROPHY SECONDARY TO DRY AMD
#563OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS
#564Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#565EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#566METHOD OF STIMULATING PROLIFERATION OF A CELL
#567Antisense oligomers and methods of using the same for treating diseases associated with the acid alpha-glucosidase gene
#568PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#569Oligonucleotide-ligand conjugates and process for their preparation
#570Compositions and methods for inhibiting nuclear receptor subfamily 1 group H member 3 (NR1H3) expression
#571COMPOSITIONS AND METHODS FOR INHIBITING KETOHEXOKINASE (KHK)
#572OLIGONUCLEOTIDES FOR TREATMENT OF ANGIOPOIETIN LIKE 4 (ANGPTL4) RELATED DISEASES
#573METHOD OF TREATING CANCER
#574Nucleic acids for inhibiting expression of TMPRSS6 and iron chelators
#575COMPOSITIONS AND METHODS FOR MODULATING ANGIOPOIETIN-LIKE 3 EXPRESSION
#576Gene editing nanocapsule and preparation method and use thereof
#577NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND CONJUGATE, PREPARATION METHOD THEREFOR AND USE THEREOF
#578COMPOUNDS AND METHODS FOR REDUCING SNCA EXPRESSION
#579COMPOSITIONS AND METHODS FOR MAKING HYBRID POLYPEPTIDES
#580COMBINATION OF HEPATITIS B VIRUS (HBV) VACCINES AND HBV-TARGETING RNAi
#581GALNAC CLUSTER PHOSPHORAMIDITE AND TARGETED THERAPEUTIC NUCLEOSIDES
#582COMPOSITIONS AND METHODS FOR INHIBITING PCSK9
#583COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#584Defined multi-conjugates oligonucleotides
#585Nucleic acids for inhibiting expression of LPA in a cell
#586COMPOUNDS AND METHODS FOR REDUCING SPDEF EXPRESSION
#587CONJUGATES AND METHODS FOR TREATING ACROMEGALY
#588MULTILAMELLAR RNA NANOPARTICLES
#589METHOD AND COMPOSITION FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#590COMPOSITIONS AND METHODS FOR THE TREATMENT OF HYPERCHOLESTEROLEMIA
#591RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING CHEMICALLY MODIFIED SHORT INTERFERING NUCLEIC ACID (SINA)
#592COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#593PRODUCTION METHOD FOR BIFURCATED LIPID-LINKED OLIGONUCLEOTIDE, AND INTERMEDIATE
#594METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#595UBE3A ANTISENSE THERAPEUTICS
#596COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#597NOVEL DNA APTAMERS AND USE THEREOF
#598EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#599REVERSIR™ compounds
#600COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TMPRSS6 GENE