109193 ⎘
Structure or type of the nucleic acid; Chemical structure; Nature of the modification Conjugate
Enhanced oligonucleotides for inhibiting RTEL1 expression
#602PEGylated synthetic KL4 peptide, Compositions and Methods Thereof
#603Phosphonate-Drug Conjugates
#604COMPOSITIONS AND METHODS FOR MODULATING TAU EXPRESSION
#605RNAi Inhibition of Alpha-ENaC Expression
#606NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#607SERPIN FAMILY F MEMBER 2 (SERPINF2) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#608OLIGONUCLEOTIDES FOR DGAT2 MODULATION
#609NUCLEIC ACID CONJUGATES AND USES THEREOF
#610COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#611Targeted inhibition using engineered oligonucleotides
#612Oral delivery of antisense conjugates targeting PCSK9
#613COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE LECT2 GENE
#614Nanoparticle to target cancer
#615RNAi agents for inhibiting expression of HIF-2 alpha (), compositions thereof, and methods of use
#616HIGH DENSITY LIPOPROTEIN BINDING PROTEIN (HDLBP/VIGILIN) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#617NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL
#618Oversubscription scheduling
#619RNA interference mediated inhibition of gene expression using short interfering nucleic acids (siNA)
#620Linkage modified oligomeric compounds and uses thereof
#621INTRACELLULAR TARGETING OF MOLECULES
#622COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#623COMPOUNDS AND METHODS FOR REDUCING KCNT1 EXPRESSION
#624Modified short interfering nucleic acid (siNA) molecules and uses thereof
#625Oligonucleotides for modulating Tau expression
#626DOUBLE-STRANDED NUCLEIC ACID INHIBITOR MOLECULES WITH SHORTENED SENSE STRANDS
#627HAIRPIN-LIKE OLIGONUCLEOTIDE-CONJUGATED SPHERICAL NUCLEIC ACID
#628Methods for treating or preventing ophthalmological conditions
#629COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
#630Modulation of prekallikrein (PKK) expression
#631Nucleic acids for inhibiting expression of LPA in a cell
#632Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use
#633NOVEL NUCLEIC ACID MODIFIERS
#634Compound for treatment of heart failure
#635OLIGONUCLEOTIDE-POLYMER MIKTOARM CONJUGATES AND METHODS OF USE
#636ANTISENSE NUCLEIC ACID TARGETING PCSK9
#637Oligonucleotides for inducing paternal UBE3A expression
#638RNA and nucleic acid carrier including the same
#639NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF PROS1 IN A CELL
#640Functionally-Modified Oligonucleotides And Subunits Thereof
#641NUCLEIC ACID CONJUGATE
#642REVERSIR TM COMPOUNDS
#643COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING
#644ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#645RNAi Inhibition of Alpha-ENaC Expression
#646PHOSPHONOACETATE GAPMER OLIGONUCLEOTIDES
#647PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS
#648Antiviral agents
#649Multi-targeted single entity conjugates
#650Methods for Oral Delivery of Oligonucleotides
#651RNAi Agents for Inhibiting Expression of Alpha-ENaC And Methods of Use
#652OLIGONUCLEOTIDES FOR HTT-1A MODULATION
#653Complement component C5 iRNA compositions and methods of use thereof
#654Products and compositions
#655APTAMER AND USE OF THE APTAMER IN THE DIAGNOSIS AND TREATMENT OF CANCER
#656DOUBLE-STRANDED NUCLEIC ACID INHIBITOR MOLECULES CONTAINING A TRILOOP
#657Compounds and methods for reducing ATXN2 expression
#658NUCLEIC ACID, COMPOSITION AND CONJUGATE CONTAINING NUCLEIC ACID, PREPARATION METHOD THEREFOR AND USE THEREOF
#659RNAi Agents for Inhibiting Expression of 17beta-HSD Type 13 (HSD17B13), Compositions Thereof, and Methods of Use
#660HBV BINDING OLIGONUCLEOTIDES AND METHODS OF USE
#661Modified double-stranded RNA agents
#662PROCESS TO INHIBIT OR ELIMINATE EOSINOPHILIC DISEASES OF THE AIRWAY AND RELATED CONDITIONS
#663EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#664RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING CHEMICALLY MODIFIED SHORT INTERFERING NUCLEIC ACID (SINA)
#665CHEMICALLY-MODIFIED RNAi CONSTRUCTS AND USES THEREOF
#666ANTISENSE OLIGONUCLEOTIDES FOR MODULATING HTRA1 EXPRESSION
#667APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#668ANTISENSE OLIGONUCLEOTIDES TARGETING CARD9
#669POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF
#670Targeting Ligands
#671METHODS FOR THE TREATMENT OF TRINUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MLH1 ACTIVITY
#672PRODUCTS AND COMPOSITIONS
#673Antisense oligomers targeting PCSK9
#674OLIGOMER-CONJUGATE COMPLEXES AND THEIR USE
#675NOVEL RNA COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL8
#676Compounds and methods for reducing prion expression
#677METHODS AND COMPOSITIONS FOR TREATING A SERPINC1-ASSOCIATED DISORDER
#678NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF C3 IN A CELL
#679POLYNUCLEOTIDE AGENTS TARGETING AMINOLEVULINIC ACID SYNTHASE-1 (ALAS1) AND USES THEREOF
#680Oligonucleotides for treatment of angiopoietin like 4 (ANGPTL4) related diseases
#681MODIFIED DOUBLE-STRANDED RNA AGENTS
#682NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#683Antisense RNA targeting PMP22 for the treatment of Charcot-Marie-Tooth 1A disease
#684Aptamers for personal health care applications
#685CXCL8 Binding Nucleic Acids
#686SiRNA conjugate, preparation method therefor and use thereof
#687RNAI AGENTS FOR HEPATITIS B VIRUS INFECTION
#688METHOD FOR REDUCING THE RISK OF A CARDIOVASCULAR EVENT WITH CONJUGATED ANTISENSE COMPOUNDS TARGETING APO(A)
#689COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRESSION
#690Compositions and methods for Editing Nucleic Acids in Cells Utilizing Oligonucleotides
#691Oligomers
#692Methods and Compositions for the ADAR-Mediated Editing of SERPINA1
#693MULTIMERIC OLIGONUCLEOTIDES HAVING DECREASED KIDNEY CLEARANCE
#694Method of delivering genes and drugs to a posterior segment of an eye
#695Methods for treating or preventing ophthalmological conditions
#696OLIGONUCLEOTIDES FOR MAPT MODULATION
#697OLIGONUCLEOTIDE MEDIATED NO-GO DECAY
#698Inhibiting angiotensinogen to attenuate aortic pathology in Marfan syndrome
#699Compositions and methods for inhibiting expression of the LECT2 gene
#700Dual-acting siRNA based modulation of C9orf72
#701KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#702Aptamer therapeutics useful in the treatment of complement-related disorders
#703MINIATURIZED HAIRPIN RNAi TRIGGERS (mxRNA) AND METHODS OF USES THEREOF
#704POLYNUCLEOTIDE AGENTS TARGETING PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) AND METHODS OF USE THEREOF
#705ANTISENSE OLIGONUCLEOTIDE (ASO) MOLECULES AND USES THEREOF FOR CORONAVIRUS DISEASES
#706SERPINA1 iRNA compositions and methods of use thereof
#707PKC INHIBITORS FOR THE TREATMENT OF SEPTIC CHOLESTASIS WITH POLYMETHINE DYE TARGETING
#708Angiotensinogen (AGT) iRNA compositions and methods of use thereof
#709RNAi agents for inhibiting expression of PNPLA3, pharmaceutical compositions thereof, and methods of use
#710CO-DELIVERY OF NUCLEIC ACIDS FOR SIMULTANEOUS SUPPRESSION AND EXPRESSION OF TARGET GENES
#711COMPOSITIONS AND AGENTS AGAINST NONALCOHOLIC STEATOHEPATITIS
#712COMPOSITIONS AND METHODS FOR THE TREATMENT OF COMPLICATIONS AND DISORDERS RELATING TO VON WILLEBRAND FACTOR
#713Method for producing dextran polymer-based, amplified nucleic acid aptamer nanoconstruct selectively capturing target molecule
#714Apolipoprotein C3 (APOC3) iRNA compositions and methods of use thereof
#715Transcriptome in vivo analysis (TIVA) and transcriptome in situ analysis (TISA)
#716Methods for treating hypercholesterolemia
#717COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTION
#718Compositions and methods for modulating PKK expression
#719Nucleic acid, composition and conjugate comprising the same, and preparation method and use thereof
#720OLIGONUCLEOTIDE-BASED PROTEOLYSIS TARGETING CHIMERA
#721Serpina1 iRNA compositions and methods of use thereof
#722RNA INTERFERENCE IN DERMAL AND FIBROTIC INDICATIONS
#723ANTISENSE OLIGONUCLEOTIDES TARGETING TIA1
#724Complement component C3 iRNA compositions and methods of use thereof
#725TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#726SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#727LINKAGE MODIFIED OLIGOMERIC COMPOUNDS
#728Methods of improving anemias by combining agents
#729Compounds and methods for increasing STMN2 expression
#730INTRACELLULAR ABSEQ
#731Oligonucleotides for modulating SCN9A expression
#732SHORT INTERFERING RNA TARGETING VARIANT C1858T OF GENE PTPN22
#733PCSK9 targeting oligonucleotides for treating hypercholesterolemia and related conditions
#734RNAi Agents And Compositions for Inhibiting Expression of Angiopoietin-Like 3 (ANGPTL3), And Methods Of Use
#735Oligonucleotide Conjugates
#736Compositions and methods for improving strand biased
#737Selective antisense compounds and uses thereof
#738General and direct method for preparing oligonucleotide-functionalized metal-organic framework nanoparticles
#739Cationic amphiphilic polymers for codelivery of hydrophobic agents and nucleic acids
#740Composition for inhibiting CTGF expression
#741STEM-LOOP COMPOSITIONS AND METHODS FOR INHIBITING INTERLEUKIN-8
#742Targeted Self-Assembly of Functionalized Carbon Nanotubes on Tumors
#743Expanding the chemical substrates for genetic code reprogramming
#744POLYNUCLEOTIDE AGENTS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12) AND METHODS OF USE THEREOF
#745COMPOSITIONS FOR MODULATING EXPRESSION OF C9ORF72 ANTISENSE TRANSCRIPT
#746Targeting PAX2 for the treatment of breast cancer
#747Compositions and methods for modulating growth hormone receptor expression
#748Nanowires/Microscale Pyramids (NWs/MPs) Complex Structure, Method for manufacturing the Same and Its Applications to Isolation of Circulating tumor cells (CTCs) and Detection of Epstein-Barr virus (EBV) DNA
#749Patatin-like phospholipase domain containing 3 (PNPLA3) iRNA compositions and methods of use thereof
#750AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#751Targeting ligands for therapeutic compounds
#752C/EBP ALPHA SARNA COMPOSITIONS AND METHODS OF USE
#753COMPOSITIONS AND USES THEREOF
#754Compositions and methods for inhibiting gene expression of Hif2alpha
#755Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#756Exon skipping compositions for treating muscular dystrophy
#757ANTI-ARID3A TREATMENTS FOR INFLAMMATORY DISORDERS
#758Compound for treatment of heart failure
#759Glucokinase (GCK) iRNA compositions and methods of use thereof
#760Antisense nucleic acid targeting PCSK9
#761POLYNUCLEOTIDE AGENTS TARGETING ANGIOTENSINOGEN (AGT) AND METHODS OF USE THEREOF
#762TMPRSS6 iRNA compositions and methods of use thereof
#763Aptamers for targeting coagulation factor XIII and uses thereof
#764PHARMACEUTICAL COMPOSITION CONTAINING COMPLEX OF CHEMICALLY-MODIFIED siRNA AND SCHIZOPHYLLAN
#765OLIGONUCLEOTIDES FOR MODULATING RTEL1 EXPRESSION
#766Selective Antisense Compounds and Uses Thereof
#767Oligonucleotides for reduction of PD-L1 expression
#768SDF-1 Binding Nucleic Acids
#769COMPOUNDS AND METHODS FOR REDUCING SPDEF EXPRESSION
#770COMPOSITIONS AND METHODS
#771Three-dimensional self-assembled nucleic acid nanoparticles and use thereof
#772Oligonucleotides for modulating Tau expression
#773POLYNUCLEOTIDE AGENTS TARGETING SERPINC1 (AT3) AND METHODS OF USE THEREOF
#774Nucleic acids for inhibiting expression of LPA in a cell
#775Methods of producing cells resistant to HIV infection
#776RNAi constructs for inhibiting ASGR1 expression and methods of use thereof
#777MicroRNA Compounds and Methods for Modulating MIR-122
#778Method of nonspecific target capture of nucleic acids
#779SMALL MOLECULE TARGETED RECRUITMENT OF A NUCLEASE TO RNA
#780Angiotensinogen (AGT) iRNA compositions and methods of use thereof
#781ANTISENSE OLIGONUCLEOTIDES TARGETING SREBP1
#782Further novel oligonucleotide-ligand conjugates
#783Compositions and methods for modulating apolipoprotein (a) expression
#784COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#785Nucleic acid linked to a trivalent glycoconjugate
#786INTEGRIN TARGETING LIGANDS AND USES THEREOF
#787Methods and compositions for inhibiting expression of LDHA
#788Oligonucleotides for modulating TMEM106B expression
#789Oligomers and oligomer conjugates
#790Conjugates of Guide RNA-Cas Protein Complex
#791CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#792CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#793Angiotensinogen (AGT) iRNA compositions and methods of use thereof
#794Modified oligonucleotides and methods of use
#795Antisense molecules and methods for treating pathologies
#796Compositions and Methods for Correcting Limb Girdle Muscular Dystrophy Type 2C Using Exon Skipping
#797Material for capturing circulating cells in the blood, method of preparation and use
#798Topical silk compositions and methods of using
#799COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#800Block copolymers
#801Methods And Compositions For Templated Assembly Of Nucleic Acid Specific Heterocompounds
#802Modified double-stranded RNA agents
#803Oligonucleotide analogues targeting human LMNA
#804Methods for modulating FMR1 expression
#805LIPOSOMAL SPHERICAL NUCLEIC ACID (SNA) CONSTRUCTS FOR SURVIVAL OF MOTOR NEURON (SMA) INHIBITORS
#806Sterol regulatory element binding protein (SREBP) chaperone (SCAP) iRNA compositions and methods of use thereof
#807Fatty acids and their use in conjugation to biomolecules
#808A DBAIT MOLECULE AGAINST ACQUIRED RESISTANCE IN THE TREATMENT OF CANCER
#809ANTISENSE OLIGONUCLEOTIDES FOR MODULATING HTRA1 EXPRESSION
#810Detection of microbial endotoxins in oral samples using aptamers
#811TMPRSS6 iRNA compositions and methods of use thereof
#812MODULATORS OF DNM2 EXPRESSION
#813Conjugated antisense compounds and their use
#814Short interfering nucleic acid (siNA) compositions
#815Nucleic acids for inhibiting expression of a target gene comprising phosphorodithioate linkages
#816Compounds and methods for reducing SNCA expression
#817RNA-editing oligonucleotides and uses thereof
#818Antisense oligonucleotides targeting ATXN3
#819Oversubscription scheduling
#820KISSPEPTIN 1 (KISS1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#821OLIGONUCLEOTIDES FOR MODULATING FNDC3B EXPRESSION
#822Nucleic acid-polypeptide compositions and uses thereof
#823POLYNUCLEOTIDE AGENTS TARGETING ANGIOTENSINOGEN (AGT) AND METHODS OF USE THEREOF
#824Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases
#825Antisense oligonucleotides for modulating the function of a T cell
#826C/EBP alpha saRNA compositions and methods of use
#827RNA nanostructures, methods of making, and uses thereof
#828Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#829Modulating apolipoprotein (a) expression
#830Nucleic acid, composition and conjugate containing same, preparation method, and use thereof
#831Antisense oligonucleotides targeting alpha-synuclein and uses thereof
#832Magnetic particle conjugates and methods of activating cell signaling
#833Oligonucleotides for inducing paternal UBE3A expression
#834COMPLEMENT COMPONENT iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#835ANTI-TNF COMPOUNDS
#836Aptamer conjugates with N-heterocyclic carbene metal complexes for targeted drug delivery
#837RNAi CONJUGATES, PARTICLES AND FORMULATIONS THEREOF
#838EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#839Multivalent oligonucleotide assemblies
#840POLYNUCLEOTIDE CONJUGATES AND USES THEREOF
#841RNAI AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#842LNA-G process
#843Compositions and methods for inhibition of HAO1 (hydroxyacid oxidase 1 (glycolate oxidase)) gene expression
#844HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#845TARGETING GLIOBLASTOMA STEM CELLS THROUGH THE TLX-TET3 AXIS
#846Xanthine dehydrogenase (XDH) IRNA compositions and methods of use thereof
#847Aptamer compositions and the use thereof
#848RNAi agents for inhibiting expression of alpha-ENaC and methods of use
#849RNAi agents and compositions for inhibiting expression of apolipoprotein C-III (APOC3)
#850Exosomal loading using hydrophobically modified oligonucleotides
#851RNAi agents and compositions for inhibiting expression of Asialoglycoprotein receptor 1
#852Methods and compositions for inhibiting expression of LDHA
#853ANTISENSE ANTIBACTERIAL COMPOUNDS AND METHODS
#854Compositions and methods for inhibiting expression of RRM2 genes
#855ANTISENSE COMPOUNDS
#856siRNA compositions that specifically down regulate expression of a variant of the PNPLA3 gene and methods of use thereof for treating a chronic liver disease
#857GALNAC DERIVATIVES
#858Single-Stranded RNAI Oligonucleotides Targeting APOC-III
#859Dynamic pharmacokinetic-modifying anchors
#860Immunostimulating-Toxic RNA In Alkaline Earth Metal Formulation
#861Complement component iRNA compositions and methods of use thereof
#862COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA
#863COMPOSITIONS AND METHODS FOR REGULATION OF GENE EXPRESSION WITH, AND DETECTION OF, FOLINIC ACID AND FOLATES
#864POLYNUCLEOTIDE AGENTS TARGETING PATATIN-LIKE PHOSPHOLIPASE DOMAIN CONTAINING 3 (PNPLA3) AND METHODS OF USE THEREOF
#865Antisense oligomers targeting PCSK9
#866Oligonucleotides for reduction of PD-L1 expression
#867Compositions for modulating expression of C9ORF72 antisense transcript
#868Method and composition for targeted delivery of therapeutic agents
#869Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof
#870COMPOSITIONS AND METHODS FOR MODULATING HBV EXPRESSION
#871SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#872Products and compositions
#873RNA LIGAND-DISPLAYING EXOSOMES FOR SPECIFIC DELIVERY OF THERAPEUTICS TO CELL BY RNA NANOTECHNOLOGY
#874STABILIZED SARNA COMPOSITIONS AND METHODS OF USE
#875METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#876Alpha-1 antitrypsin (AAT) RNAi agents, compositions including AAT RNAi agents, and methods of use
#877Nucleic acid-loaded unit polyion complex
#878REFILLABLE DRUG DELIVERY DEVICES AND METHODS OF USE THEREOF
#879PKLR inhibition in the treatment of NAFLD and HCC
#880COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#881Brush polymer-assisted compaction of oligonucleotides
#882Organic compositions to treat EPAS1-related diseases
#883COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#884Oligonucleotide compounds for treatment of preeclampsia and other angiogenic disorders
#885Methods for inhibition of HAO1 (hydroxyacid oxidase 1 (glycolate oxidase)) gene expression
#886Compositions and methods for the treatment of complications and disorders relating to Von Willebrand Factor
#887RNAi inhibition of alpha-ENaC expression
#888COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#889ANTISENSE OLIGONUCLEOTIDES FOR MODULATING HTRA1 EXPRESSION
#890Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for treating hepatitis B infection
#891Gene correction of Pompe disease and other autosomal recessive disorders via RNA-guided nucleases
#892Enzymatic replacement therapy and antisense therapy for Pompe disease
#893Compositions and methods for modulating growth hormone receptor expression
#894Modified oligonucleotides targeting SNPs
#895Functionally-modified oligonucleotides and subunits thereof
#896POLYNUCLEOTIDE AGENTS TARGETING SERPINC1 (AT3) AND METHODS OF USE THEREOF
#897Methods and compositions for managing vascular conditions
#898Products and compositions
#899CO-DELIVERY OF NUCLEIC ACIDS FOR SIMULTANEOUS SUPPRESSION AND EXPRESSION OF TARGET GENES
#900Twist signaling inhibitor compositions and methods of using the same