109236 ⎘
Production; Biochemical production, i.e. in a transformed host cell Specially adapted vectors
MALTOSE DEPENDENT DEGRONS, MALTOSE-RESPONSIVE PROMOTERS, STABILIZATION CONSTRUCTS, AND THEIR USE IN PRODUCTION OF NON-CATABOLIC COMPOUNDS
#2RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITING EXPRESSION OF DYSTROPHIA MYOTONICA PROTEIN KINASE AND/OR INTERFERING WITH A TRINUCLEOTIDE REPEAT EXPANSION IN THE 3' UNTRANSLATED REGION OF THE DMPK GENE
#3ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#4BIDIRECTIONAL MULTI-ENZYMATIC SCAFFOLDS FOR BIOSYNTHESIZING CANNABINOIDS
#5COMPOSITIONS AND METHODS FOR MUSCLE DISORDERS
#6GENE THERAPY FOR AUTOSOMAL DOMINANT DISEASES
#7INSECT CELLS AND METHODS FOR ENGINEERING THE SAME
#8ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#9COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#10HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#11METHODS OF PRODUCING CELLS RESISTANT TO HIV INFECTION
#12MODIFIED U6 PROMOTER SYSTEM FOR TISSUE SPECIFIC EXPRESSION
#13COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#14MODIFIED AAV CONSTRUCTS AND USES THEREOF
#15CRISPR/CAS9-BASED COMPOSITIONS AND METHODS FOR TREATING RETINAL DEGENERATIONS
#16RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DUX4
#17CRISPR TRANSIENT EXPRESSION CONSTRUCT (CTEC)
#18HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#19VECTORS
#20COMPOSITIONS AND METHODS FOR TREATING CANCER AND BIOMARKERS TO DETECT CANCER STEM CELL REPROGRAMMING AND PROGRESSION
#21COMPOSITIONS AND METHODS FOR TREATING CEP290 ASSOCIATED DISEASE
#22PRE-IMMUNIZATION AND IMMUNOTHERAPY
#23PRE-IMMUNIZATION AND IMMUNOTHERAPY
#24AAV TREATMENT OF HUNTINGTON’S DISEASE
#25RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING AMYOTROPHIC LATERAL SCLEROSIS
#26ENGINEERED VIRAL VECTOR REDUCES INDUCTION OF INFLAMMATORY AND IMMUNE RESPONSES
#27COMPOSITIONS AND METHODS FOR TREATING BETA-HEMOGLOBINOPATHIES
#28VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#29COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#30miRNA, and Derivative Thereof and Use Thereof
#31USE OF NOVEL MIRNA-BINDING SITE CASSETTES FOR ANTIGEN-PRESENTING CELL DETARGETING OF TRANSGENE EXPRESSION BY RAAV GENE THERAPY
#32Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
#33TRANSGENE EXPRESSION SYSTEM
#34TARGETING PEPTIDES FOR DIRECTING ADENO-ASSOCIATED VIRUSES (AAVs)
#35METHODS AND COMPOSITIONS FOR THE ACTIVATION OF GAMMA-DELTA T-CELLS
#36BIDIRECTIONAL MULTI-ENZYMATIC SCAFFOLDS FOR BIOSYNTHESIZING CANNABINOIDS
#37REAL-TIME CELLULAR THERMAL SHIFT ASSAY (RT-CETSA) FOR RESEARCH AND DRUG DISCOVERY
#38HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#39ENHANCEMENT OF THE PRODUCTION OF ADENOIDVIRUS-BASED GENETRANSFER VECTORS
#40Compositions and Methods for Treating Huntington's Disease and Related Disorders
#41ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#42RECOMBINANT AAV VECTORS WITH ALTERED IMMUNOGENCITY AND METHODS OF MAKING THE SAME
#43RNAI INDUCED HUNTINGTIN GENE SUPPRESSION
#44ONCOLYTIC VIRAL VECTORS AND USES THEREOF
#45REAGENTS FOR TREATMENT OF HEPATITIS B VIRUS (HBV) INFECTION AND USE THEREOF
#46Modified U6 promoter system for tissue specific expression
#47POTATO TRANSFORMATION VECTORS
#48MICRORNA-7 COMPOSITIONS FOR PROMOTING FUNCTIONAL RECOVERY FOLLOWING SPINAL CORD INJURY AND METHODS OF USE THEREOF
#49NOVEL PRECURSOR MIRNA AND APPLICATION THEREOF IN TUMOR TREATMENT
#50Recombinant Adeno-Associated Virus Delivery of Exon 2-Targeted U7SNRNA Polynucleotide Constructs
#51MODULAR, CELL-FREE PROTEIN EXPRESSION VECTORS TO ACCELERATE BIOLOGICAL DESIGN IN CELLS
#52Adeno-Associated Virus Vector Delivery of Microrna-29 to Treat Muscular Dystrophy
#53NUCLEIC ACID COMPOSITIONS
#54XYLANASE MUTANT HAVING IMPROVED SPECIFIC ACTIVITY
#55GENE VECTOR
#56GENE EDITING USING A MODIFIED CLOSED-ENDED DNA (CEDNA)
#57GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#58COMBINED TRANSGENE AND INTRON-DERIVED MIRNA THERAPY FOR TREATMENT OF SCA1
#59SYNTHESIS OF THE FUCOSYLATED OLIGOSACCHARIDE LNFP-V
#60FILAMENTOUS FUNGAL EXPRESSION SYSTEM
#61Recombinant virus products and methods for inducing DUX4 exon skipping
#62VECTORS AND COMPOSITIONS FOR TREATING HEMOGLOBINOPATHIES
#63Use of novel miRNA-binding site cassettes for antigen-presenting cell detargeting of transgene expression by rAAV gene therapy vectors
#64METHODS FOR CREATING INTEGRATION-FREE, VIRUS-FREE, EXOGENOUS ONCOGENE-FREE IPS CELLS AND COMPOSITIONS FOR USE IN SUCH METHODS
#65VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF PF-ILD AND IPF
#66Thermostable CAS9 nucleases
#67RETROVIRAL VECTOR HAVING IMMUNE-STIMULATING ACTIVITY
#68AAV-CAS13D VECTORS AND USES THEREOF
#69VIRAL VECTORS FOR THE TREATMENT OF DIABETES
#70TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS AND DISORDERS ASSOCIATED WITH THE SPINAL CORD
#71METHODS AND MATERIALS FOR ACTIVATING AN INTERNAL RIBOSOME ENTRY SITE IN EXON 5 OF THE DMD GENE
#72METHODS AND COMPOSITIONS FOR ALLELE SPECIFIC GENE EDITING
#73PARAVOVIRAL VECTORS AND METHODS OF MAKING AND USE THEREOF
#74RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF MYOTILIN
#75CRISPR GUIDE-RNA EXPRESSION STRATEGIES FOR MULTIPLEX GENOME ENGINEERING
#76Reagents for treatment of oculopharyngeal muscular dystrophy (OPMD) and use thereof
#77Gene therapy for retinitis pigmentosa
#78RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITING EXPRESSION OF DYSTROPHIA MYOTONICA PROTEIN KINASE AND/OR INTERFERING WITH A TRINUCLEOTIDE REPEAT EXPANSION IN THE 3' UNTRANSLATED REGION OF THE DMPK GENE
#79AAV treatment of Huntington's disease
#80Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
#81Anti-angiogenic miRNA therapeutics for inhibiting corneal neovascularization
#82RNA MEDIATED GENE REGULATING METHODS
#83Splice inhibiting oligonucleotides
#84Compositions and methods for treating beta-hemoglobinopathies
#85Modified AAV constructs and uses thereof
#86Thermostable Cas9 nucleases
#87HIV pre-immunization and immunotherapy
#88AAV VECTORS FOR TREATMENT OF DOMINANT RETINITIS PIGMENTOSA
#89RECOMBINANT AAV VECTORS USEFUL FOR REDUCING IMMUNITY AGAINST TRANSGENE PRODUCTS
#90HAEMATOPOIETIC STEM CELL-GENE THERAPY FOR WISKOTT-ALDRICH SYNDROME
#91Compositions of Asymmetric Interfering RNA and Uses Thereof
#92METHODS AND COMPOSITIONS FOR GENETICALLY MANIPULATING GENES AND CELLS
#93MULTIPLEXED SHRNAS AND USES THEREOF
#94GENE THERAPIES FOR NEURODEGENERATIVE DISEASES
#95Method for generating a gene editing vector with fixed guide RNA pairs
#96DOWN-REGULATING GENE EXPRESSION IN INSECT PLANTS
#97GENOME ENGINEERING PRIMARY MONOCYTES
#98RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#99MALTOSE DEPENDENT DEGRONS, MALTOSE-RESPONSIVE PROMOTERS, STABILIZATION CONSTRUCTS, AND THEIR USE IN PRODUCTION OF NON-CATABOLIC COMPOUNDS
#100DIRECTED EVOLUTION
#101Isolation of novel AAV's and uses thereof
#102METHODS FOR DETERMINING THE PRESENCE OR RISK OF DEVELOPING FACIOSCAPULOHUMERAL DYSTROPHY (FSHD)
#103COMPOSITIONS AND METHODS FOR MAKING ENGINEERED T CELLS
#104CRISPR-Based Synthetic Gene Circuits as Next Generation Gene Therapy of Inner Ear
#105Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
#106Oligonucleotide therapy for Leber congenital amaurosis
#107Methods of producing cells resistant to HIV infection
#108SHRNA EXPRESSION CASSETTE, POLYNUCLEOTIDE SEQUENCE CARRYING SAME, AND APPLICATION THEREOF
#109Use of MIR101 or MIR128 in the treatment of seizure disorders
#110CRISPR TRANSIENT EXPRESSION CONSTRUCT (CTEC)
#111GENE THERAPEUTIC FOR THE TREATMENT OF HIV AND USES THEREOF
#112Methods and compositions for the activation of gamma-delta T-cells
#113MALTOSE DEPENDENT DEGRONS, MALTOSE-RESPONSIVE PROMOTERS, STABILIZATION CONSTRUCTS, AND THEIR USE IN PRODUCTION OF NON-CATABOLIC COMPOUNDS
#114AAV-based treatment of cholesterol-related disorders
#115H-1 PV EXPRESSING RNAI EFFECTORS TARGETING CDK9
#116COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#117COMPOSITIONS AND METHODS FOR CORRECTING DYSTROPHIN MUTATIONS IN HUMAN CARDIOMYOCYTES
#118ANTISENSE OLIGONUCLEOTIDES FOR THE TREATMENT OF LEBER CONGENITAL AMAUROSIS
#119RECOMBINANT INSECT VECTORS AND METHODS OF USE
#120RNAi induced huntingtin gene suppression
#121Compositions and Methods for Inducing an Enhanced Immune Response Using Poxvirus Vectors
#122Compositions and methods for the expression of CRISPR guide RNAs using the H1 promoter
#123METHODS AND COMPOSITIONS FOR POLYMERASE II (POL-II) BASED GUIDE RNA EXPRESSION
#124EXON DELETION CORRECTION OF DUCHENNE MUSCULAR DYSTROPHY MUTATIONS IN THE DYSTROPHIN ACTIN BINDING DOMAIN 1 USING CRISPR GENOME EDITING
#125Splice inhibiting oligonucleotides
#126Bidirectional multi-enzymatic scaffolds for biosynthesizing cannabinoids
#127COMPOSITION AND METHOD OF USING MIR-302 PRECURSORS AS ANTI-CANCER DRUGS FOR TREATING HUMAN LUNG CANCER
#128Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
#129Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
#130Oncolytic viral vectors and uses thereof
#131DOWN-REGULATING GENE EXPRESSION IN INSECT PLANTS
#132Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
#133HIV pre-immunization and immunotherapy
#134Vectors and compositions for treating hemoglobinopathies
#135AAV treatment of Huntington's disease
#136CRISPR/CAS9-BASED COMPOSITIONS AND METHODS FOR TREATING RETINAL DEGENERATIONS
#137Compositions of asymmetric interfering RNA and uses thereof
#138Oligonucleotide therapy for Leber Congenital Amaurosis
#139Compositions of asymmetric interfering RNA and uses thereof
#140Methods for RNA promoter identification
#141Gene therapy for retinitis pigmentosa
#142RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#143Cell culture methods involving HDAC inhibitors or rep proteins
#144Methods and compositions for the activation of gamma-delta T-cells
#145Gene vector
#146Compositions and methods for the expression of CRISPR guide RNAS using the H1 promoter
#147Thermostable Cas9 nucleases
#148Exosome delivery system
#149OPTIMIZED STRATEGY FOR EXON SKIPPING MODIFICATIONS USING CRISPR/CAS9 WITH TRIPLE GUIDE SEQUENCES
#150Reagents for treatment of hepatitis B virus (HBV) infection and use thereof
#151Highly efficient and tunable system for the incorporation of unnatural amino acids into proteins in
#152Methods and compositions for multiplex RNA guided genome editing and other RNA technologies
#153Reagents for treatment of oculopharyngeal muscular dystrophy (OPMD) and use thereof
#154Thermostable CAS9 nucleases
#155RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#156METHODS AND COMPOSITIONS FOR GENETICALLY MANIPULATING GENES AND CELLS
#157Methods for creating integration-free, virus-free, exogenous oncogene-free IPS cells and compositions for use in such methods
#158Compositions and methods comprising improvements of CRISPR guide RNAS using the H1 promoter
#159NUCLEIC ACID CONSTRUCTS INCLUDING A TXNIP PROMOTER FOR THE TREATMENT OF DISEASE
#160HOMEOSTATIC REGULATION OF L-DOPA BIOSYNTHESIS
#161Methods and compositions for in vivo induction of pancreatic beta cell formation
#162Recombinant virus products and methods for inhibition of expression of DUX4
#163METHODS AND COMPOSITIONS FOR T-RNA BASED GUIDE RNA EXPRESSION
#164Method for modifying genes
#165Compositions and methods for mitochondrial genome editing
#166E. COLI MEDIATED siRNA SILENCING OF AVIAN INFLUENZA IN CHICKENS
#167Isolation of novel AAV's and uses thereof
#168Viral vectors for treating Parkinson's disease
#169Novel Paratransgenic System for the Biocontrol of Disease-Transmitting Mosquitos
#170RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#171Recombinant adeno-associated virus delivery of exon 2-targeted U7SNRNA polynucleotide constructs
#172MicroRNA-200 based approaches for modulating bone formation inhibition and bone regeneration
#173AAV delivery of shRNA for treatment of pancreatic cancer
#174Recombinant virus products and methods for inhibition of expression of myotilin
#175CTLA-4-targeting trans-splicing ribozyme for delivery of chimeric antigen receptor, and use thereof
#176HIV pre-immunization and immunotherapy
#177siRNA knocking down human PD-1 and recombinant expression CAR-T vector and their construction methods and applications
#178HIV pre-immunization and immunotherapy
#179Anti-aging transgenic Caenorhabditis elegans
#180CRISPR-CAS system for a filamentous fungal host cell
#181AAV-based treatment of cholesterol-related disorders
#182Human induced pluripotent stem cells for high efficiency genetic engineering
#183Engineered viral vector reduces induction of inflammatory and immune responses
#184Compositions and methods for treating CEP290 associated disease
#185Use of MIR101 or MIR128 in the treatment of seizure disorders
#186COMPOSITIONS AND METHODS RELATED TO THERAPEUTIC CELL SYSTEMS EXPRESSING EXOGENOUS RNA
#187Compositions and methods for treating Huntington's disease
#188Inhibitory RNA-based therapeutics targeting ANLN for cancer treatment
#189RNAi induced huntingtin gene suppression
#190Modified U6 promoter system for tissue specific expression
#191Adeno-associated virus vector delivery of microrna-29 to treat muscular dystrophy
#192Cancer therapy
#193Compositions and methods for treating beta-hemoglobinopathies
#194AAV vectors for treatment of dominant retinitis pigmentosa
#195System for the biocontrol of disease-transmitting mosquitoes and their eggs using horizontally transferable symbiotic bacteria to deliver pathogen specific interfering RNA polynucleotides
#196In-vitro induction of adult stem cell expansion and derivation
#197Conditional CRISPR sgRNA expression
#198Methods and compositions for the activation of gamma-delta T-cells
#199Therapeutic for treatment of diseases including the central nervous system
#200Adeno-associated virus vector delivery of microRNA-29 and micro-dystrophin to treat muscular dystrophy
#201Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy
#202Compositions and methods for treating Huntington's disease and related disorders
#203Anti-angiogenic miRNA therapeutics for inhibiting corneal neovascularization
#204Method of producing cells resistant to HIV infection
#205Compositions and Methods to Treat Latent Viral Infections
#206Recombinant virus products and methods for inducing DUX4 exon skipping
#207Nucleic acid molecule, expression cassette, expression vector, eukaryotic host cell, induction method of RNA interference in eukaryotic host and use of the nucleic acid molecule in therapy of diseases induced by expansion of trinucleotide CAG repeats
#208Treatment of heart disease by inhibtion of the action of muscle A-kinase anchoring protein (mAKAP)
#209Compositions and methods for the expression of CRISPR guide RNAs using the H1 promoter
#210Oncolytic viral vectors and uses thereof
#211Culicinae Mosquito TRA-2 RNA Interference Technique to Genetically Produce Maleness Population
#212Enhanced protein expression and methods thereof
#213Methods and compositions for integration defective lentiviral vectors
#214AGE-RELATED MACULAR DEGENERATION TREATMENT
#215Modified AAV constructs and uses thereof
#216Linalool composition and method of producing therefor
#217Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
#218Methods for modulating KLHL1 levels, methods for modulating current activity in T-type calcium channels, molecules therefor, and methods for identifying molecules therefor
#219RNA and method for specifically activating human RSPO2 gene with CRISPR-Cas9 and application thereof
#220Viral vectors for the treatment of diabetes
#221Delivery, use and therapeutic applications of the CRISPR-cas systems and compositions for modeling mutations in leukocytes
#222Precursor miRNA and applications in tumor therapy thereof
#223Compositions and methods for treating leukemia
#224Paratransgenic system for the biocontrol of disease-transmitting mosquitos
#225NOVEL PRECURSOR MIRNA AND APPLICATION THEREOF IN TUMOR TREATMENT
#226Antibody Fusion Protein and Preparation Method and Use Thereof
#227Compositions and methods for the expression of CRISPR guide RNAs using the H1 promoter
#228Cancer specific-splicing ribozyme and use thereof
#229Maltose dependent degrons, maltose-responsive promoters, stabilization constructs, and their use in production of non-catabolic compounds
#230Vectors
#231Maltose dependent degrons, maltose-responsive promoters, stabilization constructs, and their use in production of non-catabolic compounds
#232Immortalised chicken embryo fibroblasts
#233Methods of delivery of transgenes for treating brain diseases
#234In vivo production of small interfering RNAs that mediate gene silencing
#235NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS OF USE THEROF
#236RNA-guided transcriptional regulation and methods of using the same for the treatment of back pain
#237Methods for RNA promoter identification
#238Down-regulating gene expression in insect plants
#239GENOME EDITING VECTORS
#240MiRNA compositions for the treatment of mature B-cell neoplasms
#241Cyanobacterial strains capable of utilizing phosphite
#242AAV treatment of Huntington's disease
#243Gene vector
#244Use and production of CHD8+/− transgenic animals with behavioral phenotypes characteristic of autism spectrum disorder
#245Identification of a 5-Gene Expression Signature Predicting Clinical Outcome of Patients with Brain Tumors
#246Replication capable rAAV vectors encoding inhibitory siRNA and methods of their use
#247Oligonucleotide therapy for leber congenital amaurosis
#248Double-stranded ribonucleic acid as control against insects
#249Reduction of off-target RNA interference toxicity
#250RNAI induced huntingtin gene suppression
#251Method of conveniently producing genetically modified non-human mammal with high efficiency
#252USE OF MICRORNA PRECURSORS AS DRUGS FOR INDUCING CD34-POSITIVE ADULT STEM CELL EXPANSION
#253ADIPOCYTE-SPECIFIC CONSTRUCTS AND METHODS FOR INHIBITING PLATELET-TYPE 12 LIPOXYGENASE EXPRESSION
#254Recombinant RNA Viruses and Uses Thereof
#255Fusarium chitin synthase gene chs3b and the use thereof
#256MicroRNA-200 based approaches for modulating bone formation inhibition and bone regeneration
#257Methods and compositions for in vivo induction of pancreatic beta cell formation
#258Methods for characterizing alternatively or aberrantly spliced mRNA isoforms
#259RNA-targeting system
#260Microrna inhibitor system and methods of use thereof
#261Adeno-associated viral vectors for treating myocilin (MYOC) glaucoma
#262Methods and compositions for use of non-coding RNA in cell culturing and selection
#263PLASMIDS COMPRISING INTERNAL RIBOSOMAL ENTRY SITES AND USES THEREOF
#264Multiplexed shRNAs and uses thereof
#265Magnetic control of gene delivery in vivo
#266Live attenuated viral vaccine created by self-attenuation with species-specific artificial MicroRNA
#267Methods and materials for activating an internal ribosome entry site in exon 5 of the DMD gene
#268Nurr1 as a genetic target for treating levodopa-induced dyskinesias in Parkinson's disease
#269Isolated oleaginous yeast
#270Retroviral vector having immune-stimulating activity
#271Composition and method of using miR-302 precursors as anti-cancer drugs for treating human lung cancer
#272Gene therapy for retinitis pigmentosa
#273Isolation of novel AAV's and uses thereof
#274Targeting peptides for directing adeno-associated viruses (AAVs)
#275Recombinant AAV vectors useful for reducing immunity against transgene products
#276Isolation of novel AAV's and uses thereof
#277Treatment of amyotrophic lateral sclerosis
#278RAAV-based compositions and methods for treating amyotrophic lateral sclerosis
#279Methods and compositions for inhibiting retinopathy of prematurity
#280SiRNA in tandem expression and uses thereof in treating chronic lymphocytic leukemia
#281Recombinant virus products and methods for inhibition of expression of DUX4
#282Method and compositions for controlling pest insects on plants by silencing genes of the chitin synthase and of the vitellogenin family, as well as alternatively by expressing the gene of a cry toxin
#283METHODS AND COMPOSITIONS FOR THE PRODUCTION OF GUIDE RNA
#284Nucleic acid molecule, expression cassette, expression vector, eukaryotic host cell, induction method of RNA interferencde in eukaryotic host and use of the nucleic acid molecule in therapy of diseases induced by expansion of trinucleotide CAG repeats
#285In vivo production of small interfering RNAs that mediate gene silencing
#286DNA vector production system
#287Recombinant virus products and methods for inhibition of expression of myotilin
#288Compositions of asymmetric interfering RNA and uses thereof
#289Methods and compositions for multiplex RNA guided genome editing and other RNA technologies
#290Use of microRNA precursors as drugs for inducing CD34-positive adult stem cell expansion
#291COMPOSITIONS AND METHODS FOR SILENCING EBOLA VIRUS GENE EXPRESSION
#292Methods for inducing cardiomyocyte proliferation
#293Use of novel monosaccharide-like glycylated sugar alcohol compositions for designing and developing anti-diabetic drugs
#294AAV-based treatment of cholesterol-related disorders
#295Effective method for specific gene silencing using artificial small RNA
#296Means and methods for the generation of mammalian producer cells for the production of recombinant proteins
#297Methods and compositions involving lincRNA and leukemia
#298Age-related macular degeneration treatment
#299Dosage compensating transgenes and cells
#300Isolation of novel AAV's and uses thereof