110536 ⎘
ssDNA viruses; Details; Parvoviridae; Dependovirus, e.g. adenoassociated viruses New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
ADENO-ASSOCIATED VIRUS VIRIONS AND METHODS OF USE THEREOF
#302MANUFACTURING METHOD OF ADENO-ASSOCIATED VIRUS, CELL, AND EXPRESSION VECTOR
#303Method for the Production of AAV
#304MODIFIED AAV CAPSIDS AND USES THEREOF
#305LYOPHILIZED NON-VIRAL DNA VECTOR COMPOSITIONS AND USES THEREOF
#306AMINO ACIDS, NUCLEOTIDES AND VECTORS EXPRESSING THE SAME AND USES THEREOF IN PREVENTING SARBECOVIRUS INFECTION
#307AAV FOR THE GENE THERAPY OF WET-AMD
#308RECOMBINANT ADENO-ASSOCIATED VIRUS HAVING VARIANT CAPSID, AND APPLICATION THEREOF
#309COMPOSITIONS AND METHODS FOR ADENO-ASSOCIATED VIRAL PRODUCTION
#310EXPRESSION CASSETTE FOR EXPRESSING GENE COMPRISING OVERLAPPING OPEN READING FRAMES IN INSECT CELL AND APPLICATION THEREOF
#311AAV VIRION ENCODING NEUROTROPHIC FACTOR AND USES THEREOF
#312Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#313GENE THERAPY FOR TREM2-ASSOCIATED DISEASES AND DISORDERS
#314COMPOSITIONS AND METHODS FOR TREATING SENSORINEURAL HEARING LOSS USING STEREOCILIN DUAL VECTOR SYSTEMS
#315DIRECT RAAV-MEDIATED IN VIVO GENE EDITING OF HEMATOPOIETIC STEM CELLS
#316AAV Capsids and Uses Thereof
#317METHODS AND COMPOSITIONS FOR GENE TRANSFER ACROSS THE VASCULATURE
#318Peptide-Modified AAV Capsid
#319NOVEL COMPOSITIONS WITH BRAIN-SPECIFIC TARGETING MOTIFS AND COMPOSITIONS CONTAINING SAME
#320G-PROTEIN-GATED-K+ CHANNEL-MEDIATED ENHANCEMENTS IN LIGHT SENSITIVITY IN ROD-CONE DYSTROPHY (RCD)
#321COMPOSITIONS AND METHODS FOR TREATMENT OF CRX-MEDIATED RETINOPATHIES
#322Recombinant Adeno-Associated Vectors For Targeted Treatment
#323CAPSID VARIANTS AND USES THEREOF
#324AAV CAPSIDS WITH INCREASED TROPISM TO BRAIN TISSUE
#325METHODS OF REDOSING GENE THERAPY VECTORS
#326METHODS FOR PRODUCING SINGLE INSECT CELL CLONES
#327ADENO-ASSOCIATED VIRAL VECTORS FOR TRANSDUCTION OF COCHLEA
#328RECOMBINANT AAVS FOR DELIVERY TO CENTRAL NERVOUS SYSTEM AND BRAIN VASCULATURE
#329TISSUE-TARGETED MODIFIED AAV CAPSIDS AND METHODS OF USE THEREOF
#330METHODS OF TREATING OCULAR DISEASES USING AAV2 VARIANTS ENCODING AFLIBERCEPT
#331RECOMBINANT HERPESVIRALES VECTOR
#332RATIONAL POLYPLOID AAV VIRIONS THAT CROSS THE BLOOD BRAIN BARRIER AND ELICIT REDUCED HUMORAL RESPONSE
#333OLIGONUCLEOTIDES TARGETING S6K1
#334AAVRH74 VECTORS FOR GENE THERAPY OF MUSCULAR DYSTROPHIES
#335COMPOSITION AND METHODS FOR THE TREATMENT OF FABRY DISEASE
#336ARSB VECTORS FOR TREATMENT OF MPS VI-ASSOCIATED BLINDNESS AND OTHER OCULAR MANIFESTATIONS
#337Compositions and Methods for Producing Recombinant AAV
#338Methods and compositions for delivery of viral vectors across the blood-brain barrier
#339METHODS AND COMPOSITIONS FOR ANTIBODY-EVADING VIRUS VECTORS
#340METHODS AND COMPOSITIONS FOR CIRCULAR RNA MOLECULES
#341CONTROLLED EXPRESSION OF VIRAL PROTEINS
#342CONTROLLED EXPRESSION OF VIRAL PROTEINS
#343COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS AND/OR VISION LOSS
#344Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#345GENE THERAPY FOR TREM2-ASSOCIATED DISEASES AND DISORDERS
#346ADENO-ASSOCIATED VIRUS VECTOR
#347ADENO-ASSOCIATED VIRUSES AND METHODS AND MATERIALS FOR MAKING AND USING ADENO-ASSOCIATED VIRUSES
#348VECTORIZED ANTI-CGRP AND ANTI-CGRPR ANTIBODIES AND ADMINISTRATION THEREOF
#349Auxotrophic Cells for Virus Production and Compositions and Methods of Making
#350AAV VECTORS TARGETING T-CELLS
#351HYBRID AAV-ANELLOVECTORS
#352Method of Increasing the Function of an AAV Vector
#353NOVEL ADENO-ASSOCIATED VIRUS (AAV) CLADE F VECTOR AND USES THEREFOR
#354METHODS AND COMPOSITIONS FOR TREATMENT OF CYSTIC FIBROSIS
#355RECOMBINANT AAVS WITH IMPROVED TROPISM AND SPECIFICITY
#356RECOMBINANT AAV1, AAV5, AND AAV6 CAPSID MUTANTS AND USES THEREOF
#357METHODS OF REGULATING ADENO-ASSOCIATED VIRUS PRODUCTION
#358MICROTUBULE DESTABILIZER ADDITIVES TO INCREASE RECOMBINANT VIRAL VECTOR TITERS
#359Adeno-associated virus compositions for targeted gene therapy
#360ADENO-ASSOCIATED VIRAL VECTOR VARIANTS
#361Self-complementary AAV vectors carrying dominant negative RhoA and methods of use to treat ocular diseases
#362AAV CAPSID PRODUCTION IN INSECT CELLS
#363Compositions and methods of treating ocular diseases
#364MUTATED ADENO-ASSOCIATED VIRAL CAPSID PROTEINS FOR CHEMICAL COUPLING OF LIGANDS, NANOPARTICLES OR DRUGS VIA THIOETHER BINDING AND PRODUCTION METHOD THEREOF
#365VIRAL VECTOR FOR THE TARGETED TRANSFER OF GENES IN THE BRAIN AND SPINAL CORD
#366Cross-species compatible adeno-associated virus compositions and methods of use thereof
#367CODON-OPTIMIZED NUCLEIC ACID ENCODING THE FIX PROTEIN
#368HELPER PLASMID AND METHOD FOR PREPARING RECOMBINANT ADENO-ASSOCIATED VIRUS
#369Cross-species compatible adeno-associated virus compositions and methods of use thereof
#370ADENO-ASSOCIATED VARIANTS, FORMULATIONS AND METHODS FOR PULMONARY DELIVERY
#371Recombinant adeno-associated virus vectors
#372ADENO-ASSOCIATED VIRUS CAPSIDS AND VECTORS
#373ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS WITH IMPROVED RETINAL TRANSDUCTION AND USES THEREOF
#374METHODS AND COMPOSITIONS FOR MODULATING THE INTERACTION BETWEEN ADENO-ASSOCIATED VIRUS (AAV) AND THE AAV RECEPTOR (AAVR) FOR ALTERED BIO-DISTRIBUTION OF AAV
#375LIGHT-CONTROLLED VIRAL TRANSDUCTION
#376AAV CAPSIDS AND VECTORS
#377Antibody-evading virus vectors
#378Antibody-evading virus vectors
#379ENGINEERED VIRAL CAPSIDS AND METHODS OF USE
#380Adenoviruses and methods for using adenoviruses
#381RECOMBINANT ADENO-ASSOCIATED VIRUSES WITH ENHANCED LIVER TROPISM AND USES THEREOF
#382NOVEL COMPOSITIONS WITH TISSUE-SPECIFIC TARGETING MOTIFS AND COMPOSITIONS CONTAINING SAME
#383VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#384METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#385VECTORS WITH MODIFIED INITIATION CODON FOR THE TRANSLATION OF AAV-REP78 USEFUL FOR PRODUCTION OF AAV
#386AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#387USE OF IRAK4 MODULATORS FOR GENE THERAPY
#388LIVER DE-TARGETED RECOMBINANT AAV CAPSID PROTEINS
#389RATIONAL POLYPLOID ADENO-ASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF DISEASE
#390COMPOSITIONS COMPRISING AAV-BINDING POLYPEPTIDES AND METHODS OF USING THE SAME
#391VECTORIZED FACTOR XII ANTIBODIES AND ADMINISTRATION THEREOF
#392EXPRESSION CASSETTE OF GENE COMPRISING OVERLAPPING OPEN READING FRAMES AND APPLICATION THEREOF IN INSECT CELL
#393ADENO-ASSOCIATED VIRUSES FOR OCULAR DELIVERY OF GENE THERAPY
#394AAV CAPSID DESIGNS
#395RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR CNS OR MUSCLE DELIVERY
#396IMPROVED ADENO-ASSOCIATED VIRUS GENE THERAPY VECTORS
#397ANTEROGRADE MONOSYNAPTIC TRANSNEURONAL TRACER SYSTEM WITH GK PROTEIN FUNCTION MANIPULATION
#398Adenoviruses and methods for using adenoviruses
#399ENGINEERED AAV VECTORS
#400METHOD OF ENGINEERING AND ISOLATING ADENO-ASSOCIATED VIRUS
#401Capsid variants and methods of using the same
#402IMPROVED DEPENDOPARVOVIRUS PRODUCTION COMPOSITIONS AND METHODS
#403Inducible AAV REP genes
#404ADENO-ASSOCIATED VIRAL VECTOR VARIANTS
#405METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#406ADENO-ASSOCIATED VIRUS FOR DELIVERY OF KH902 (CONBERCEPT) AND USES THEREOF
#407INACTIVE TELOMERASE, ADENOVIRUS ASSOCIATED VIRUS AND ARTIFICIAL MRNA HAVING SAME AND USE THEREOF
#408TREATMENT OF RPE65-ASSOCIATED EYE DISEASES AND DISORDERS
#409NOVEL ENGINEERED CAPSID SEROTYPE OF RECOMBINANT ADENO-ASSOCIATED VIRAL VECTOR WITH ENHANCED TRANSDUCTION EFFICIENCY AND WIDESPREAD DISTRIBUTION IN THE BRAIN
#410Compositions and Methods of Treatment
#411COMPOSITIONS AND METHODS FOR REDUCING OCULAR NEOVASCULARIZATION
#412NOVEL ADENO-ASSOCIATED VIRUS CAPSID PROTEINS
#413ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#414CELL LINE FOR USE IN PRODUCING RECOMBINANT ADENOVIRUSES
#415MODIFIED ADENO-ASSOCIATED VIRUS VECTORS THAT EVADE NEUTRALIZING ANTIBODIES AND USES THEREOF
#416Compositions and methods for delivery of AAV
#417ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED EXPRESSION LEVELS
#418CELL CULTURE MEDIUM FOR USE IN PRODUCING GENE THERAPY PRODUCTS IN BIOREACTORS
#419COMPOSITION AND METHOD
#420METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#421NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#422Methods for using transcription-dependent directed evolution of AAV capsids
#423Methods for using transcription-dependent directed evolution of AAV capsids
#424Methods of predicting ancestral virus sequences and uses thereof
#425GENE THERAPIES FOR LYSOSOMAL DISORDERS
#426Adeno-associated virus variant capsids and methods of use thereof
#427GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS IIIA
#428ADENOVIRUS VECTORS AND METHODS FOR USING ADENOVIRUS VECTORS
#429CELL LINES FOR RECOMBINANT AAV PRODUCTION AND AAV-IMPLEMENTED PROTEIN PRODUCTION
#430RECOMBINANT AAV VECTORS FOR TREATING NERVOUS SYSTEM DISEASES
#431METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#432USE OF CIRCUTRN IN PREPARATION OF DRUG FOR TREATING HEART FAILURE, RECOMBINANT VECTOR, AND DRUG FOR TREATING HEART FAILURE
#433AAV VECTORS TARGETED TO THE CENTRAL NERVOUS SYSTEM
#434Adeno-associated variants, formulations and methods for pulmonary delivery
#435METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV2.5 VECTOR
#436Methods and compositions for antibody-evading virus vectors
#437Method for Engineering Novel Hybrid AAV Capsids Through Hyper Variable Regions Swapping
#438COMPOSITIONS AND METHODS FOR REDUCING REVERSE PACKAGING OF CAP AND REP SEQUENCES IN RECOMBINANT AAV
#439GENE THERAPY FOR OCULAR DISORDERS
#440BIFUNCTIONAL BRIDGING COMPOSITIONS FOR VIRAL TRANSDUCTION
#441ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#442CODON-OPTIMIZED NUCLEIC ACID ENCODING SMN1 PROTEIN
#443ADENO-ASSOCIATED VIRUS VECTOR AND USE THEREOF
#444Treatments for retinal disease
#445COMPOSITIONS FOR TREATING FRIEDREICH’S ATAXIA
#446COMPOSITIONS USEFUL IN TREATMENT OF KRABBE DISEASE
#447METHODS FOR ANALYZING AAV CAPSID PROTEINS
#448METHODS AND COMPOSITIONS FOR CIRCULAR RNA MOLECULES
#449REDIRECTION OF TROPISM OF AAV CAPSIDS
#450Adeno-associated virus vector variants for high efficiency genome editing and methods thereof
#451ENGINEERED CENTRAL NERVOUS SYSTEM COMPOSITIONS
#452METHODS FOR USING TRANSCRIPTION-DEPENDENT DIRECTED EVOLUTION OF AAV CAPSIDS
#453GENE THERAPY OF NIEMANN-PICK DISEASE TYPE C
#454DISEASE CORRECTION BY DELIVERY OF AAV8 VECTORS EXPRESSING CODON OPTIMIZED NAGLU
#455AAV PRODUCTION STRATEGY USING A CELL LINE EXPRESSING AN INDUCIBLE REP GENE
#456METHODS AND COMPOSITIONS FOR THE PURIFICATION OF ADENO-ASSOCIATED VIRUS
#457PEPTIDES HAVING SPECIFICITY FOR THE LUNGS
#458Restrictive inverted terminal repeats for viral vectors
#459METHODS AND COMPOSITIONS FOR PRODUCTION OF RECOMBINANT ADENO-ASSOCIATED VIRUSES
#460G-PROTEIN-GATED-K+ CHANNEL-MEDIATED ENHANCEMENTS IN LIGHT SENSITIVITY IN ROD-CONE DYSTROPHY (RCD)
#461CROSS-SPECIES COMPATIBLE ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF
#462AAV CAPSIDS VARIANTS AND USES THEREOF
#463CAPSID-MODIFIED RAAV VECTOR COMPOSITIONS AND METHODS THEREFOR
#464REDIRECTION OF TROPISM OF AAV CAPSIDS
#465High-transduction-efficiency rAAV vectors, compositions, and methods of use
#466PREPARATION METHOD AND SYSTEM FOR RECOMBINANT ADENO-ASSOCIATED VIRUS, AND RECOMBINANT BACMID
#467RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS IN PLANTS
#468AAV CAPSID VARIANTS
#469Viral vector particle based on AA V2 for gene therapy
#470PROSTATE TARGETING ADENO-ASSOCIATED VIRUS SEROTYPE VECTORS
#471AAV capsids identified by in vivo library selection
#472A PROCESS FOR PRODUCING A PLURALITY OF SUMOYLATION TARGET-SITE MODIFIED AAV VECTOR AND PRODUCT THEREOF
#473Dual helper plasmid
#474Methods and compositions for delivery of immunotherapy agents across the blood-brain barrier to treat brain cancer
#475COMPOSITIONS AND METHODS FOR ENHANCING VISUAL FUNCTION
#476NOVEL AAV3B VARIANTS THAT TARGET HUMAN HEPATOCYTES IN THE LIVER OF HUMANIZED MICE
#477ADENO ASSOCIATED VIRAL VECTORS
#478Compositions and methods for identifying RNA binding polypeptide targets
#479ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF
#480ADENO-ASSOCIATED VIRUS PACKAGING SYSTEMS
#481AAV CAPSID-PROMOTER INTERACTIONS AND CELL SELECTIVE GENE EXPRESSION
#482AAV3B VARIANTS WITH IMPROVED PRODUCTION YIELD AND LIVER TROPISM
#483SYNTHETIC ADENO-ASSOCIATED VIRUS INVERTED TERMINAL REPEATS AND METHODS OF THEIR USE AS PROMOTERS
#484VIRAL CAPSID POLYPEPTIDES
#485Treatments for retinal disease
#486METHODS AND COMPOSITIONS FOR MODULATING THE INTERACTION BETWEEN ADENO-ASSOCIATED VIRUS (AAV) AND THE AAV RECEPTOR (AAVR) FOR ALTERED BIO-DISTRIBUTION OF AAV
#487EFFECTIVE DOSAGES OF AN ADENOVIRAL-BASED BIOLOGICAL DELIVERY AND EXPRESSION SYSTEM FOR USE IN THE TREATMENT OF OSTEOARTHRITIS IN HUMANS, AND COMPOSITIONS COMPRISING THE SAME
#488NOVEL AAV VARIANT
#489Adeno-associated virus capsid proteins
#490VIRAL CAPSID POLYPEPTIDES
#491ENHANCED DELIVERY OF VIRAL PARTICLES TO THE STRIATUM AND CORTEX
#492Compositions and methods of treatment
#493ON-BIPOLAR CELL-SPECIFIC PROMOTERS FOR OCULAR GENE DELIVERY
#494VECTORS AND GENE THERAPY FOR TREATING CORNELIA DE LANGE SYNDROME
#495Method for delivering RNA to neurons to treat herpes infections
#496LACTAM-MODIFIED ADENO-ASSOCIATED VIRUS VECTORS
#497Adeno-Associated Viral Vectors for Crossing the Human Blood Brain Barrier
#498METHODS AND AAV VECTORS FOR IN VIVO TRANSDUCTION
#499ENHANCED PLATFORMS FOR UNNATURAL AMINO ACID INCORPORATION IN MAMMALIAN CELLS
#500KCNV2 variants and their use
#501VACCINE AND METHOD FOR TREATING CANCER
#502TARGETING DELTAFOSB FOR TREATMENT OF DYSKINESIA
#503ADENO-ASSOCIATED VIRUS VIRIONS WITH VARIANT CAPSID AND METHODS OF USE THEREOF
#504ADENO-ASSOCIATED VIRUSES AND THEIR USES FOR INNER EAR THERAPY
#505AAVRH74 VECTORS FOR GENE THERAPY OF MUSCULAR DYSTROPHIES
#506ENGINEERED MUSCLE TARGETING COMPOSITIONS
#507Adeno-associated virus virions with variant capsid and methods of use thereof
#508Adeno-associated virus virions with variant capsid and methods of use thereof
#509ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#510CHARACTERIZATION OF GENE THERAPY VIRAL PARTICLES USING SIZE EXCLUSION CHROMATOGRAPHY AND MULTI-ANGLE LIGHT SCATTERING TECHNOLOGIES
#511IMPROVED PRODUCTION OF RECOMBINANT AAV USING EMBRYONATED AVIAN EGGS
#512RECOMBINANT HERPESVIRALES VECTOR
#513A PROCESS FOR PRODUCING A PLURALITY OF NEDDYLATION SITE MODIFIED AAV VECTORS
#514ISOLATED MODIFIED VP1 CAPSID PROTEIN OF AAV5
#515VIRAL PARTICLES FOR USE IN TREATING SYNUCLEINOPATHIES SUCH AS PARKINSON'S DISEASES BY GENE THERAPY
#516PROGRAMMABLE DNA BASE EDITING BY NME2CAS9-DEAMINASE FUSION PROTEINS
#517MODIFIED ADENO-ASSOCIATED VIRUS (AAV) PARTICLES FOR GENE THERAPY
#518CHEMICALLY-MODIFIED ADENO-ASSOCIATED VIRUS
#519Methods and materials for producing recombinant viruses in eukaryotic microalgae
#520AAV CAPSID VARIANTS FOR GENE THERAPY
#521AAV VARIANTS WITH ENHANCED TROPISM
#522New Adeno-Associated Virus (AAV) Variants and Uses Thereof for Gene Therapy
#523Adeno-associated virus virions for treatment of epilepsy
#524ENHANCED TRANSDUCTION OF AAV VECTORS ENCODING MICRORNAS
#525Modified AAV Capsid Proteins for Treatment of Arthritic Disease
#526ADENO-ASSOCIATED VIRUS PURIFICATION METHODS
#527Modified AAV capsid proteins and uses thereof
#528ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#529NOVEL AAV LIBRARY
#530AAV VECTORS PRODUCED BY INSECT CELLS COMPRISING REP52 AND REP78 CODING SEQUENCES WITH DIFFERENTIAL CODON BIASES
#531Adeno-associated virus variant capsids and methods of use thereof
#532NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#533Adeno-Associated Virus Virions with Variant Capsid and Methods of Use Thereof
#534Engineered muscle targeting compositions
#535PRODUCTION OF VECTORS USING PHAGE ORIGIN OF REPLICATION
#536COMPOSITIONS AND METHODS FOR PRODUCING ADENO-ASSOCIATED VIRAL VECTORS
#537COMPOSITIONS AND METHODS FOR TREATMENT OF CYSTIC FIBROSIS
#538MODIFIED VIRAL PARTICLES AND USES THEREOF
#539EXPRESSION VECTOR AGAINST SEVERE ACUTE RESPIRATORY SYNDROME VIRUS SARS-COV-2
#540MINIGENE THERAPY
#541RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS TO TARGET MEDULLARY THYROID CARCINOMA
#542AAV MUTANT THAT EFFICIENTLY INFECTS SUPPORTING CELLS
#543ENGINEERED MUSCLE TARGETING COMPOSITIONS
#544COMPOSITIONS USEFUL IN TREATMENT OF METACHROMATIC LEUKODYSTROPHY
#545Modified AAV capsids and uses thereof
#546VIRUS COMPOSITIONS WITH ENHANCED SPECIFICITY IN THE BRAIN
#547NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#548NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
#549Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#550NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#551ENGINEERED ADENO-ASSOCIATED (AAV) VECTORS FOR TRANSGENE EXPRESSION
#552Closed-ended linear duplex DNA for non-viral gene transfer
#553METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV2.5 VECTOR
#554RAAV WITH CHEMICALLY MODIFIED CAPSID
#555RECOMBINANT ADENO-ASSOCIATED VIRUSES AND USES THEREOF
#556MUTATED ADENO-ASSOCIATED VIRUS CAPSID PROTEINS, AAV PARTICLE COMPRISING THE SAME AND LIVER DIRECTED AAV VECTOR GENE THERAPY
#557FASL IMMUNOMODULATORY GENE THERAPY COMPOSITIONS AND METHODS FOR USE
#558PLASMID SYSTEM
#559GENE THERAPY METHODS
#560SYSTEMS FOR EVOLVED ADENO-ASSOCIATED VIRUSES (AAVS) FOR TARGETED DELIVERY
#561METHODS AND SYSTEMS OF PCR-BASED RECOMBINANT ADENO-ASSOCIATED VIRUS MANUFACTURE
#562Methods and compositions for dual glycan binding AAV2.5 vector
#563HIGHLY EFFICIENT TRANSDUCTION AND LATERAL SPREAD IN THE RETINA BY A NOVEL AAV VIRUS ENHANCED BY RATIONAL DESIGN
#564MODULATION OF REP PROTEIN ACTIVITY IN CLOSED-ENDED DNA (CEDNA) PRODUCTION
#565ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR TARGETED GENE THERAPY
#566ADENO-ASSOCIATED VIRUS VECTOR
#567Selective recovery
#568ADENO-ASSOCIATED VIRUSES AND THEIR USES FOR INNER EAR THERAPY
#569Methods and compositions for circular RNA molecules
#570RECOMBINANT ADENO-ASSOCIATED VIRAL VECTOR FOR GENE DELIVERY
#571Methods and compositions for antibody-evading virus vectors
#572Methods and compositions for delivery of agents across the blood-brain barrier
#573COMPOSITIONS AND METHODS FOR THE TREATMENT OF DEGENERATIVE OCULAR DISEASES
#574RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS
#575Adenovirus vectors and methods for using adenovirus vectors
#576AAV capsids with increased tropism to brain tissue
#577Method of detecting and/or identifying adeno-associated virus (AAV) sequences and isolating novel sequences identified thereby
#578Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses therefor
#579Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#580PLASMID FREE AAV VECTOR PRODUCING CELL LINES
#581Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses therefor
#582ADENO-ASSOCIATED VIRUS VARIANTS AND METHODS OF USE THEREOF
#583METHODS OF PREDICTING ANCESTRAL VIRUS SEQUENCES AND USES THEREOF
#584AAVrh.10 variants with host antibody escape capabilities and altered tissue targeting properties
#585AAV VIRIONS WITH DECREASED IMMUNOREACTIVITY AND USES THEREFOR
#586Materials and methods for delivering nucleic acids to cochlear and vestibular cells
#587EXPRESSION VECTORS FOR LARGE-SCALE PRODUCTION OF rAAV IN THE BACULOVIRUS/Sf9 SYSTEM
#588Adeno-associated variants, formulations and methods for pulmonary delivery
#589NUCLEIC ACID MOLECULES AND METHODS FOR AAV VECTOR SELECTION
#590COMPOSITIONS AND METHODS FOR INTRAVITREAL DELIVERY OF POLYNUCLEOTIDES TO RETINAL CONES
#591Anti-angiogenic miRNA therapeutics for inhibiting corneal neovascularization
#592REDIRECTION OF TROPISM OF AAV CAPSIDS
#593Adeno-associated virus variant capsids and methods of use thereof
#594RECOMBINANT ADENO-ASSOCIATED VECTORS
#595Adeno-associated virus virions with variant capsids and methods of use thereof
#596Antibody-evading virus vectors
#597COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
#598Virus vectors for targeting ophthalmic tissues
#599MODIFIED AAV CAPSID POLYPEPTIDES FOR TREATMENT OF MUSCULAR DISEASES
#600ENGINEERED AAV CAPSIDS WITH INCREASED TROPISM AND AAV VECTORS COMPRISING THE ENGINEERED CAPSIDS AND METHODS OF MAKING AND USING SAME