110536 ⎘
ssDNA viruses; Details; Parvoviridae; Dependovirus, e.g. adenoassociated viruses New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
MODIFIED CPG DINUCLEOTIDES FOR RECOMBINANT VIRAL VECTOR PRODUCTION
#2METHOD OF REDUCING CST FLUCTUATION IN NEOVASCULAR AMD BY A RECOMBINANT ADENO-ASSOCIATED VIRUS
#3LACTAM-MODIFIED ADENO-ASSOCIATED VIRUS VECTORS
#4HYBRID AAV VECTOR ENHANCING TRANSGENE EXPRESSION IN THE LIVER
#5METHOD FOR THE PRODUCTION OF RECOMBINANT AAV PARTICLE PREPARATIONS
#6ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED BRAIN ENRICHMENT AND LOW LIVER ENRICHMENT
#7GENE THERAPY VECTORS FOR THE EXPRESSION OF PREPRODYNORPHIN VARIANTS FOR THE TREATMENT OF EPILEPSY
#8AAV PARTICLES COMPRISING LIVER-TROPIC CAPSID PROTEIN AND ACID ALPHA-GLUCOSIDASE AND USE TO TREAT POMPE DISEASE
#9GENE THERAPY FOR PRADER WILLI SYNDROME
#10GENE INTRODUCTION METHOD, GENE THERAPY METHOD, AND TISSUE REGENERATION METHOD
#11ENGINEERED MUSCLE TARGETING COMPOSITIONS
#12ADENO-ASSOCIATED VIRUS VARIANT AND USE THEREOF
#13PLASMID SYSTEM
#14Polynucleotides for use in AAV production
#15COMPOSITIONS AND METHODS FOR TREATING DUCHENNE MUSCULAR DYSTROPHY
#16ADENO-ASSOCIATED VIRUS VARIANT
#17AAV CAPSID VARIANTS AND USES THEREOF
#18rAAV PRODUCTION IN INSECT CELLS
#19ADENO-ASSOCIATED VIRUS (AAV) DIRECTED ANTIOXIDATIVE GENE THERAPY FOR THE PREVENTION, AMELIORATION, AND/OR TREATMENT OF HEARING LOSS
#20CAPSID VARIANTS AND METHODS OF USING THE SAME
#21NOVEL DUAL HELPER PLASMID
#22RECOMBINANT AAV VECTORS FOR TREATING PROTEINOPATHIES IN CENTRAL NERVOUS SYSTEM
#23AAV CAPSID VARIANTS AND USES THEREOF
#24CAPSID POLYPEPTIDES AND METHODS OF USE THEREOF
#25COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED GENE TARGETING FOR THE TREATMENT OF GENETIC DISORDERS IN ADULT PATIENTS
#26ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#27ENGINEERED MUSCLE TARGETING COMPOSITIONS
#28RECOMBINANT AAVS WITH IMPROVED TROPISM AND SPECIFICITY
#29BBB interacting capsids
#30RECOMBINANT ADENO-ASSOCIATED VIRUSES AND USES THEREOF
#31HYBRID AAV CAPSID AND USES THEREOF
#32ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS WITH IMPROVED RETINAL TRANSDUCTION AND USES THEREOF
#33NOVEL ADENO-ASSOCIATED VIRUS (AAV) VECTORS, AAV VECTORS HAVING REDUCED CAPSID DEAMIDATION AND USES THEREFOR
#34Variant AAV and Compositions, Methods and Uses for Gene Transfer to Cells, Organs and Tissues
#35ENHANCED DELIVERY OF VIRAL PARTICLES TO THE STRIATUM AND CORTEX
#36AAV CAPSID PROTEINS HAVING MUTATIONS IN THE VP1 REGION
#37VARIANT AAV CAPSID POLYPEPTIDES TARGETING THE EYE
#38ADENO-ASSOCIATED VIRUS CAPSID HAVING TISSUE TROPISM AND USE THEREOF
#39NOVEL AAV3B CAPSID VARIANTS WITH ENHANCED HEPATOCYTE TROPISM
#40REDIRECTION OF TROPISM OF AAV CAPSIDS
#41AAV VECTORS PRODUCED BY INSECT CELLS COMPRISING REP52 AND REP78 CODING SEQUENCES WITH DIFFERENTIAL CODON BIASES
#42VECTORIZED ANTI-COMPLEMENT ANTIBODIES AND COMPLEMENT AGENTS AND ADMINISTRATION THEREOF
#43METHODS FOR CHARACTERIZING A PROTEIN
#44SPLIT RECOMBINASES HAVING INDUCIBLE RECOMBINASE ACTIVITY
#45SELECTED ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED BRAIN, SPINAL CORD, AND/OR HEART EXPRESSION LEVELS
#46CAPSID POLYPEPTIDES AND METHODS OF USE THEREOF
#47Novel AAV rep ORFs and Rep polypeptides
#48GENETIC CIRCUITS
#49RECOMBINANT AAV HAVING AAV CLADE D AND CLADE E CAPSIDS AND COMPOSITIONS CONTAINING SAME
#50ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#51COMPOSITIONS AND METHODS FOR TREATING NON-AGE-ASSOCIATED HEARING IMPAIRMENT IN A HUMAN SUBJECT
#52MUSCLE-SPECIFIC REGULATORY CASSETTES
#53Adeno-Associated Virus Variant Capsids with Improved Lung Tropism and Uses Thereof
#54System for High-Level rAAV Production
#55AAV-MEDIATED DELIVERY OF RGS10 TO MICROGLIA
#56ADENO-ASSOCIATED VIRUS GENE THERAPY PRODUCTS AND METHODS
#57GENE THERAPIES FOR TREATMENT OF INFANTILE NEUROAXONAL DYSTROPHY
#58ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#59MODIFIED ADENO-ASSOCIATED VIRUS CAPSID PROTEINS AND METHODS THEREOF
#60GENE THERAPY FOR FAM161A-ASSOCIATED RETINOPATHIES AND OTHER CILIOPATHIES
#61VIRAL VECTOR GENOME ENCODING AN INSULIN FUSION PROTEIN
#62WNT-MODULATING GENE SILENCERS AS BONE ANABOLIC THERAPY FOR OSTEOPOROSIS AND CRITICAL-SIZED BONE DEFECT
#63CAPSID VARIANTS AND METHODS OF USING THE SAME
#64ENGINEERED ADENO-ASSOCIATED VIRUS CAPSIDS
#65AAV CAPSID VARIANTS AND USES THEREOF
#66GENE THERAPY COMPOSITIONS AND METHODS FOR TREATING DISEASES OF THE RETINA
#67AAV2 VARIANTS AND USES THEREOF
#68ADENO-ASSOCIATED VIRUS FORMULATIONS
#69Gene constructs for silencing alpha-synuclein and uses thereof
#70AAV-BASED GENE THERAPY FOR HEREDITARY ANTITHROMBIN DEFICIENCY
#71FUSION TYPE ADENO-ASSOCIATED VIRUS AND USE THEREOF
#72MUSCLE TROPIC RAAV
#73GENE THERAPY FOR TREATING MITOCHONDRIAL STRESS
#74VECTOR-BASED GENE THERAPY FOR ELONGATOR ACETYLTRANSFERASE COMPLEX SUBUNIT 1 (ELP1)
#75MINIGENE THERAPY
#76NOVEL AAV CAPSID-MODIFIED STRAIN AND USE THEREOF
#77NOVEL RECOMBINANT AAV VP2 FUSION POLYPEPTIDES
#78CAPSID VARIANTS AND METHODS OF USING THE SAME
#79CAPSID VARIANTS AND METHODS OF USING THE SAME
#80DELIVERING GENES TO THE BRAIN ENDOTHELIUM TO TREAT LYSOSOMAL STORAGE DISORDER-DERIVED NEUROPATHOLOGY
#81AAV VECTOR ENCODING DIAMINE OXIDASE AND USES THEREOF
#82IMMUNE TOLERANCE INDUCTION TO VIRAL CAPSIDS
#83COMPOUNDS FOR IMPROVEMENT OF VIRAL PRODUCTION
#84BACULOVIRUS EXPRESSION SYSTEM
#85ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT AND DECREASED LIVER ENRICHMENT
#86NOVEL SYSTEM FOR THE DETECTION AND QUANTIFICATION OF ANTI-AAV NEUTRALIZING ANTIBODIES
#87GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING LOSS
#88ADENO-ASSOCIATED VIRUS VIRION FOR TREATING ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#89CHEMICALLY-MODIFIED ADENO-ASSOCIATED VIRUSES
#90ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL CELLS
#91VECTORIZED LANADELUMAB AND ADMINISTRATION THEREOF
#92VIRAL CAPSID PROTEINS WITH SPECIFICITY TO HEART TISSUE CELLS
#93MUTANT OF ADENO-ASSOCIATED VIRUS AND USE THEREOF
#94EFFECTIVELY PACKAGING HIGH-QUALITY RAAV VECTORS BY MINICIRCLE DUAL TRANSFECTION
#95AAV VECTORS FOR RETINAL AND CNS GENE THERAPY
#96AAV VECTORS ENCODING SOD1-TARGETING ARTIFICIAL MIRNAS (AMI-RNA)
#97CAPSID VARIANTS AND METHODS OF USING THE SAME
#98AAV5 CAPSID WITH NON-CANONICAL AMINO ACID INCORPORATION AND USES THEREOF
#99CAPSID VARIANTS AND USES THEREOF
#100MUTANT OF ADENO-ASSOCIATED VIRUS AND USE THEREOF
#101COMPOSITIONS USEFUL IN TREATMENT OF METACHROMATIC LEUKODYSTROPHY
#102ADENO-ASSOCIATED VIRUS CAPSIDS
#103COMPOSITIONS FOR RESTORING MECP2 GENE FUNCTION AND METHODS OF USE THEREOF
#104RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR FOR TREATMENT OF IRON-ACCUMULATING NEURODEGENERATIVE DISEASES
#105ADENO-ASSOCIATED VIRAL VECTORS FOR TARGETING BRAIN MICROVASCULATURE
#106METHOD FOR EXPRESSING A MUSCLE-SPECIFIC GENE AND CASSETTES FOR SAME
#107Compositions and Methods for Enhanced Production of Adeno-Associated Virus
#108MUTANT OF ADENO-ASSOCIATED VIRUS AND USE THEREOF
#109ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#110RECOMBINANT AAV VECTORS AND USE THEREOF
#111Insect cell-produced high potency AAV vectors with CNS-tropism
#112COMPOSITIONS AND METHODS FOR THE TREATMENT OF HER2 POSITIVE CANCER
#113CLOSED-ENDED LINEAR DUPLEX DNA FOR NON-VIRAL GENE TRANSFER
#114METHODS FOR PROCESSING AND ANALYZING VIRUS CAPSID PROTEINS
#115SELECTED AAV COMPOSITIONS HAVING PREFERRED BRAIN ENRICHMENT
#116COMPOSITIONS AND METHODS FOR TREATING CHRONIC PAIN AND FOR RETROGRADE TRANSDUCTION OF NEURONS
#117MUTANT OF ADENO-ASSOCIATED VIRUS CAPSID PROTEIN
#118HYBRID AAV CAPSIDS
#119FULLY-HUMAN POST-TRANSLATIONALLY MODIFIED ANTIBODY THERAPEUTICS
#120ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY
#121Producer Cell Having Low Levels of VA-RNA
#122IMMORTALIZED CELLS FOR PRODUCTION OF BIOPRODUCTS, METHODS OF PRODUCING BIOPRODUCTS WITH AN IMMORTALIZED CELL, AND METHODS OF MAKING IMMORTALIZED CELLS FOR PRODUCTION OF BIOPRODUCTS
#123AAV CAPSID PROTEINS FOR NUCLEIC ACID TRANFER
#124GENE THERAPY
#125CAPSID VARIANTS AND METHODS OF USING THE SAME
#126MODIFIED VIRUSES AND VIRAL PARTICLES, METHODS OF MAKING, AND USES THEREOF
#127ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT AND/OR HEART ENRICHMENT
#128CAPSIDS FOR PLAKOPHILLIN-2 GENE THERAPY
#129OPTIMIZATION OF HEK293 SUSPENSION PLATFORM FOR IMPROVED rAAV TITERS
#130CAPSID VARIANTS AND METHODS OF USING THE SAME
#131GENE THERAPY FOR TREATING AN OCULAR DISEASE
#132ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#133PRODUCTION OF VIRUS VECTOR PLASMID IN BACILLUS SUBTILIS
#134DEGRON FUSION CONSTRUCTS
#135METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
#136INTEGRATIVE PLASMID
#137AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS WITH THE TRANSFERRIN RECEPTOR
#138AAV CAPSID VARIANTS AND USES THEREOF
#139AAV VECTOR ENCODING ANTI-VEGF-A AND ANG-2 BISPECIFIC ANTIBODY
#140GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING LOSS
#141ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RETINAL REGIONS
#142AAV CAPSID VARIANTS AND USES THEREOF
#143METHODS AND COMPOSITIONS FOR DELIVERY OF VIRAL VECTORS ACROSS THE BLOOD-BRAIN BARRIER
#144ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL GANGLION CELLS AND/OR RETINAL PIGMENT EPITHELIUM CELLS
#145TRANSCRIPTION-DEPENDENT DIRECTED EVOLUTION OF AAV CAPSIDS HAVING ENHANCED TROPISM
#146FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION
#147EFFICIENT SYSTEM FOR PRODUCING ADENO-ASSOCIATED VIRUS (AAV) VECTOR
#148ARTIFICIAL microRNAs TARGETING TAU
#149NOVEL AAV CAPSIDS FOR TARGETING NERVOUS SYSTEM AND USES THEREOF
#150Compositions Comprising Adeno-Associated Virus Chimera Capsid Proteins and Methods of Using the Same
#151GENE THERAPY FOR GLAUCOMA
#152METHODS OF RAAV PACKAGING
#153CONJUGATION OF ADENO-ASSOCIATED VIRUSES
#154SELECTED AAV COMPOSITIONS HAVING PREFERRED BRAIN ENRICHMENT
#155ADENO-ASSOCIATED VIRAL VECTOR CAPSIDS WITH IMPROVED TISSUE TROPISM
#156EXPRESSION SYSTEM FOR THE TREATMENT OF CANCER
#157ADENO-ASSOCIATED VIRAL VECTOR COMPOSITIONS AND METHODS OF PROMOTING MUSCLE REGENERATION
#158METHODS AND COMPOSITIONS FOR TARGETED GENE TRANSFER
#159METHOD OF INTRODUCING NUCLEIC ACID INTO CELL AND APPLICATION THEREOF
#160ADENOVIRUS VECTORS AND METHODS FOR USING ADENOVIRUS VECTORS
#161METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#162RECOMBINANT AAV VECTORS AND USES THEREOF
#163RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR CNS TROPIC DELIVERY
#164ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR TARGETED GENE THERAPY
#165GENE THERAPY FOR THE TREATMENT OF HT1
#166METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
#167CpG REDUCED FACTOR VIII VARIANTS, COMPOSITIONS AND METHODS AND USES FOR TREATMENT OF HEMOSTASIS DISORDERS
#168AAV VECTORS FOR DELIVERY OF GLP-1 RECEPTOR AGONIST FUSIONS
#169GENE THERAPEUTICS FOR TREATING BONE DISORDERS
#170THERAPEUTIC FACTORS FOR THE TREATMENT OF POLYQ DISEASES
#171ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS AND METHODS OF USE THEREOF
#172COVALENTLY SURFACE MODIFIED ADENO-ASSOCIATED VIRUS PRODUCTION BY IN VITRO CONJUGATION, AND PURIFICATION OF COVALENTLY SURFACE MODIFIED ADENO-ASSOCIATED VIRUS
#173IMPROVED CELL LINES AND METHODS FOR THE PRODUCTION OF ADENO-ASSOCIATED VECTORS
#174INTEGRATIVE PLASMID
#175CHIMERIC LUNG TROPIC AAV CAPSIDS
#176CHIMERIC NEUROTROPIC AAV CAPSIDS
#177AAV CAPSID VARIANTS AND USES THEREOF
#178ADENO-ASSOCIATED VIRUS VECTOR VARIANTS FOR HIGH EFFICIENCY GENOME EDITING AND METHODS THEREOF
#179ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#180METHOD OF OBTAINING A MODIFIED ADENO-ASSOCIATED VIRUS CAPSID
#181METHODS OF TREATING GAUCHER DISEASE AND GBA-PARKINSON’S DISEASE
#182METHODS OF TREATING NEURODEGENERATIVE DISORDERS
#183TEMPLATED MUTAGENESIS AND NUCLEIC ACID SYNTHESIS
#184Deamidation Depleted Adeno-Associated Virus Product
#185METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS
#186AAV CAPSIDS FOR IMPROVED HEART TRANSDUCTION AND DETARGETING OF LIVER
#187GENE THERAPY FOR THE TREATMENT OF WILSON'S DISEASE
#188METHODS OF TREATING OCULAR NEOVASCULAR DISEASES USING AAV2 VARIANTS ENCODING AFLIBERCEPT
#189ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF
#190COMPOSITIONS AND METHODS FOR TREATING SIALIDOSIS
#191METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS
#192Isolated modified capsid protein VP1 from adeno-associated virus serotype 5 (AAV5), capsid and vector based thereon
#193CAPSID
#194AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#195PRODUCTION AND PURIFICATION OF COVALENTLY SURFACE MODIFIED ADENO-ASSOCIATED VIRUS
#196RECOMBINANT AAV CAPSID PROTEINS
#197GENE THERAPY FOR GENETIC HEARING LOSS
#198SYSTEMS OF SINGLE-CELL LABELING AND METHODS OF USING THE SAME
#199MODIFIED CPG DINUCLEOTIDES FOR RECOMBINANT VIRAL VECTOR PRODUCTION
#200MODIFIED VECTOR, CONSTRUCTION METHOD, AND APPLICATION OF MODIFIED AAV-8 SEROTYPE FOR GENE TARGETING AND EXPRESSION
#201OPTIMIZED AAV-BASED VACCINE
#202MODIFIED AAV CAPSID PROTEIN AND USE THEREOF
#203MODIFIED ADENO-ASSOCIATED VIRUS VECTOR
#204AAV TRANSFER PLASMIDS
#205ANTIBODY-EVADING VIRUS VECTORS
#206EXPRESSION CASSETTES FOR TREATING EPILEPSY AND NEUROPATHIC PAIN
#207ENGINEERED MUSCLE TARGETING COMPOSITIONS
#208ADENO-ASSOCIATED VIRUS VECTORS
#209VECTOR CONSTRUCTS FOR DELIVERY OF NUCLEIC ACIDS ENCODING THERAPEUTIC ANTI-IGF-1R ANTIBODIES AND METHODS OF USING THE SAME
#210ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
#211AAV5 CAPSID VARIANTS
#212TRANSGENE CASSETTES DESIGNED TO EXPRESS THE HUMAN CODON-OPTIMIZED GENE FMR1
#213ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
#214METHODS AND COMPOSITIONS FOR DELIVERY OF IMMUNOTHERAPY AGENTS ACROSS THE BLOOD-BRAIN BARRIER TO TREAT BRAIN CANCER
#215ENGINEERED VIRAL CAPSIDS WITH INCREASED STABILITY AND METHODS OF USE THEREOF
#216CAPSID VARIANTS AND METHODS OF USING THE SAME
#217RECOMBINANT AAV VECTORS FOR TREATING GLUTARIC ACIDURIA TYPE I
#218RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV) GENOME AND SINGLE-POLARITY RAAV VECTOR PACKAGED THEREBY
#219Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#220ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF
#221ENGINEERED MUSCLE TARGETING COMPOSITIONS
#222MODIFIED VIRAL CAPSIDS
#223COMPOSITONS AND METHODS FOR THE TREATMENT OF NEUROLOGICAL DISORDERS RELATED TO GLUCOSYLCERAMIDASE BETA DEFICIENCY
#224ENGINEERED MUSCLE TARGETING COMPOSITIONS
#225HIGH EFFICIENCY LIBRARY-IDENTIFIED AAV VECTORS
#226ADENOVIRUSES AND METHODS FOR USING ADENOVIRUSES
#227Adeno-Associated-Virus Rep Sequences, Vectors and Viruses
#228FUNCTIONAL AAV CAPSIDS FOR INTRAVITREAL ADMINISTRATION
#229RECOMBINANT AAV CAPSID PROTEINS
#230PRODUCTION OF RECOMBINANT AAV VECTORS FOR TREATING MUSCULAR DYSTROPHY
#231Inducible AAV REP genes
#232GENE THERAPY FOR SPINAL MUSCULAR ATROPHY
#233KCNV2 Variants and Their Use
#234AAV CAPSID VARIANTS AND USES THEREOF
#235VIRAL ADAPTORS AND USES THEREOF
#236ENGINEERED CENTRAL NERVOUS SYSTEM COMPOSITIONS
#237AAV CAPSID VARIANTS AND USES THEREOF
#238ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED HEART AND SKELETAL MUSCLE ENRICHMENT
#239RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR TARGETED DELIVERY
#240CAPSID VARIANTS AND METHODS OF USING THE SAME
#241CAPSID VARIANTS AND METHODS OF USING THE SAME
#242MODIFIED AAV CAPSID POLYPEPTIDES AND VECTORS
#243GENE THERAPY FOR SPINAL MUSCULAR ATROPHY
#244ENGINEERED MUSCLE AND CENTRAL NERVOUS SYSTEM COMPOSITIONS
#245AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GALACTOSIDASE AND THEIR USE TO TREAT FABRY DISEASE
#246NOVEL METHODS OF USING ADENO-ASSOCIATED VIRUS 11 (AAV11)
#247CAPSID VARIANTS AND METHODS OF USING THE SAME
#248METHODS FOR PURIFICATION OF RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS FOR GENE THERAPY
#249ENGINEERED CARDIAC MUSCLE COMPOSITIONS
#250RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEPTIDES
#251AAVRH74 PARTICLES FOR GENE THERAPY OF MUSCLE DISEASE
#252PRODUCTION OF VIRUS VECTOR PLASMID IN BACILLUS SUBTILIS
#253METHODS AND COMPOSITIONS TO SPREAD PROTEIN CARGOES ACROSS MULTI-NUCLEATED CELLS
#254AAV8 CAPSID VARIANTS WITH ENHANCED LIVER TARGETING
#255TARGETING MOIETIES PROMOTING TRANSDUCTION OF CENTRAL NERVOUS SYSTEM CELLS AND TISSUES AND METHODS OF USE
#256NOVEL AAV CAPSIDS AND COMPOSITIONS CONTAINING SAME
#257AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#258RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS
#259VIRUS COMPOSITIONS TO EFFICIENTLY TARGET THE NERVOUS SYSTEM AND THE LUNGS
#260AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#261AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
#262RECOMBINANT AAV CONSTRUCTS FOR INCREASED TRANSGENE EXPRESSION
#263AAV capsid variants and uses thereof
#264Adeno-associated virus vectors modified to bind High-Density Lipoprotein
#265AAV Vectors Targeted to Oligodendrocytes
#266Genetically Engineered Eukaryotic Cells and Cell Lines and Uses Thereof
#267METHODS AND MATERIALS FOR PRODUCING RECOMBINANT VIRUSES IN EUKARYOTIC MICROALGAE
#268CAPSID VARIANTS AND METHODS OF USING THE SAME
#269ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF
#270SELF-INACTIVATING VECTORS FOR GENE EDITING
#271STABLE PRODUCTION SYSTEMS FOR ADENO-ASSOCIATED VIRUS PRODUCTION
#272MODIFIED AAV CAPSIDS AND VECTORS
#273ISOLATED MODIFIED AAV9 CAPSID PROTEIN VP1
#274VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IGK SIGNAL SEQUENCE
#275ENGINEERING AAV VECTORS WITH IMPROVED CNS TARGETING
#276ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS AND USE FOR INHIBITING ANGIOGENESIS
#277ADENO-ASSOCIATED VIRUS CAPSID
#278METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS
#279ENGINEERED TARGETING COMPOSITIONS FOR ENDOTHELIAL CELLS OF THE CENTRAL NERVOUS SYSTEM VASCULATURE AND METHODS OF USE THEREOF
#280AAV Vectors
#281FUSION PROTEINS COMPRISING A PROTEIN WITH PHASE BEHAVIOR
#282Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism
#283ADENO-ASSOCIATED VIRUS CAPSID PROTEINS
#284PHARMACEUTICAL COMPOSITIONS CONTAINING ADENO-ASSOCIATED VIRAL VECTOR
#285MODIFIED AAV CAPSIDS AND USES THEREOF
#286NOVEL AAV SEROTYPES DERIVED FROM A LIBRARY SCREEN
#287VIRAL DELIVERY OF A SIALIDASE TO TREAT CANCER
#288COMPOSITIONS AND METHODS FOR ACHIEVING HIGH LEVELS OF TRANSDUCTION IN HUMAN LIVER CELLS
#289BACULOVIRUS EXPRESSION SYSTEM
#290CAPSID VARIANTS AND METHODS OF USING THE SAME
#291COMPOSITIONS AND METHODS FOR FORMATION AND SECRETION OF EXTRACELLULAR VESICLES AND AAV PARTICLES
#292REPLICATION-COMPETENT ADENOVIRUS TYPE 4 SARS-COV-2 VACCINES AND THEIR USE
#293Improved lysis procedures
#294AAV VECTOR VARIANTS FOR OCULAR GENE DELIVERY
#295COMPOSITION AND METHOD FOR TREATING HEMOPHILIA B
#296CETYLTRIMETHYLAMMONIUM BROMIDE (CTAB) AS A LYSIS AND FLOCCULATION REAGENT IN GENE THERAPY DOWNSTREAM PROCESSES
#297CAPSID VARIANTS AND METHODS OF USING THE SAME
#298CAPSID VARIANTS AND METHODS OF USING THE SAME
#299METHODS AND COMPOSITIONS FOR TREATING OCULAR DISEASES AND DISORDERS
#300ADENO-ASSOCIATED VIRUS VIRIONS AND METHODS OF USE THEREOF