112297 ⎘
Vector systems having a special element relevant for transcription being a stuffer
CONSTRUCTS COMPRISING NEURONAL VIABILITY FACTORS AND USES THEREOF
#2ADENO-ASSOCIATED VIRUS VECTORS FOR TREATMENT OF RETT SYNDROME
#3RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS
#4NOVEL AAV VECTORS AND METHODS AND USES THEREOF
#5VECTORS COMPRISING STUFFER POLYNUCLEOTIDE SEQUENCES
#6ADENO-ASSOCIATED VIRUS VECTORS FOR TREATMENT OF RETT SYNDROME
#7RECOMBINASE COMPOSITIONS AND METHODS OF USE
#8THERAPEUTIC ADENO-ASSOCIATED VIRUS COMPRISING LIVER-SPECIFIC PROMOTERS FOR TREATING POMPE DISEASE AND LYSOSOMAL DISORDERS
#9NUCLEIC ACID MOLECULES CONTAINING SPACERS AND METHODS OF USE THEREOF
#10RECOMBINANT VECTORS COMPRISING ARYLSULFATASE A AND THEIR USES IN STEM CELL THERAPY FOR THE TREATMENT OF METACHROMATIC LEUKODYSTROPHY
#11Adeno-associated virus vectors for treatment of Rett syndrome
#12NUCLEIC ACID MOLECULES CONTAINING SPACERS AND METHODS OF USE THEREOF
#13VARIANT RNAi AGAINST ALPHA-SYNUCLEIN
#14Recombinant adeno-associated viral vectors
#15PRODUCTION OF VIRAL VECTORS
#16Nucleic acid molecules containing spacers and methods of use thereof
#17Nucleic acid molecules containing spacers outside ITR
#18MODIFIED ADENO-ASSOCIATED VIRUS VECTOR COMPOSITIONS
#19Production of viral vectors
#20Synthetic genes and genetic constructs
#21Methods and compositions relating to improved lentiviral vector production systems
#22Modified adeno-associated virus vector compositions
#23Vectors for transgene expression
#24Production of viral vectors
#25Control of gene expression
#26Synthetic genes and genetic constructs
#27CONTROL OF GENE EXPRESSION
#28Synthetic genes and genetic constructs
#29TREATMENT AND PREVENTION OF INFLUENZA
#30Production of viral vectors
#31Packaging cells for recombinant adenovirus
#32Method of adenoviral vector synthesis
#33Methods and compositions relating to improved lentiviral vector production systems
#34Self-rearranging DNA vectors
#35Gutless adenovirus vector and the construction method thereof
#36Adenovirus vectors comprising meganuclease-type endonucleases, and related systems
#37Packaging cells for recombinant adenovirus
#38Episomal expression system
#39Cells expressing recombinase useful for adenovirus vector production and control of gene expression
#40Control of gene expression
#41Control of gene expression
#42Methods of unidirectional, site-specific integration into a genome, compositions and kits for practicing the same
#43Use of aminoglycoside resistance gene
#44Packaging systems for human recombinant adenovirus to be used in gene therapy
#45Adenoviral vector system
#46Pseudotyped lentiviral vectors and uses thereof