112328 ⎘
Vectors comprising a special translation-regulating system being a specific part of the splice mechanism, e.g. donor, acceptor for trans-splicing, e.g. polypyrimidine tract, branch point splicing
SPLIT PRIME EDITORS
#2COMPOSITIONS AND METHODS FOR EXPRESSING OTOFERLIN
#3INTRON FRAGMENTS
#4VECTORS
#5RNA Trans-Splicing Molecule
#6COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS AND/OR VISION LOSS
#7CRISPR/CAS9-MEDIATED MEANS AND METHODS FOR CELL REPROGRAMMING
#8USE OF A SPLIT dCAS FUSION PROTEIN SYSTEM FOR EPIGENETIC EDITING
#9COMPOSITIONS AND METHODS FOR USING ALTERNATIVE SPLICING TO CONTROL SPECIFICITY OF GENE THERAPY
#10SYSTEMS AND USES THEREOF FOR CREATING SYNTHETIC TRANSCRIPTIONAL LOGIC 'AND' GATES BASED ON PRE-mRNA TRANS-SPLICING
#11COMPOSITIONS AND METHODS FOR HIGH-EFFICIENCY RECOMBINATION OF RNA MOLECULES
#12METHODS AND COMPOSITIONS FOR BARCODING NUCLEIC ACID LIBRARIES AND CELL POPULATIONS
#13COMPOSITIONS AND METHODS FOR TREATING NEUROCOGNITIVE DISORDERS
#14Intron fragments
#15MULTIPLE VECTOR SYSTEM AND USES THEREOF
#16DUAL-AAV VECTOR-BASED SYSTEMS AND METHODS FOR DELIVERING OVERSIZED GENES TO MAMMALIAN CELLS
#17Expression Constructs and Methods for Expressing Polypeptides in Eukaryotic Cells
#18Dual-AAV vector-based systems and methods for delivering oversized genes to mammalian cells
#19Hybrid dual recombinant AAV vector systems for gene therapy
#20Cyclized cytokines and method for producing same
#21Vectors
#22Expression Constructs and Methods for Expressing Polypeptides in Eukaryotic Cells
#23Effective delivery of large genes by dual AAV vectors
#24Recombinant adenovirus with increased safety and anticancer activities, and use thereof
#25EXPRESSION CONSTRUCTS AND METHODS FOR EXPRESSING POLYPEPTIDES IN EUKARYOTIC CELLS
#26Dual-AAV vector-based systems and methods for delivering oversized genes to mammalian cells
#27Promoters exhibiting endothelial cell specificity and methods of using same
#28Mini-intronic plasmid vectors
#29Nucleic acid molecules and methods for exchanging exon(s) by transsplicing
#30Pre-MRNA trans-splicing molecule (RTM) molecules and their uses
#31NUCLEIC ACID MOLECULES AND METHODS FOR EXCHANGING EXON(S) BY TRANSSPLICING
#32Promoters exhibiting endothelial cell specificity and methods of using same
#33RECOMBINANT ADENOVIRUS COMPRISING TISSUE-SPECIFIC PROMOTER AND TUMOR-TARGETING TRANS-SPLICING RIBOZYME AND USES THEREOF
#34PROMOTERS EXHIBITING ENDOTHELIAL CELL SPECIFICITY AND METHODS OF USING SAME
#35Methods and Compositions for Regulated Expressions of Nucleic Acid at Post-Transcriptional Level
#36Promoters exhibiting endothelial cell specificity and methods of using same
#37TRANS-SPLICING MEDIATED PHOTODYNAMIC THERAPY
#38Generation of tumor-free embryonic stem-like pluripotent cells using inducible recombinant RNA agents
#39Addition of transgenes into adenoviral vectors
#40Methods and compositions for use in spliceosome mediated RNA trans-splicing
#41Process of producing environmentally safe transgenic organisms
#42Methods and compositions for use in spliceosome mediated RNA trans-splicing in plants
#43Gene regulation with aptamer and modulator complexes for gene therapy
#44Cytomegalovirus Intron A fragments
#45Promoters exhibiting endothelial cell specificity and methods of using same
#46Cytomegalovirus Intron A fragments