108937 ⎘
Enzymes; Proenzymes; Compositions thereof ; Processes for preparing, activating, inhibiting, separating or purifying enzymes; Hydrolases (3) acting on ester bonds (3.1) Ribonucleases RNAses, DNAses
COMPOSITIONS AND METHODS FOR THE TARGETING OF PCSK9
#2702RING NUCLEASE
#2703HTRA1 MODULATION FOR TREATMENT OF AMD
#2704COMPOSITIONS AND METHODS FOR MODIFYING A TARGET NUCLEIC ACID
#2705METHODS OF EDITING SINGLE NUCLEOTIDE POLYMORPHISM USING PROGRAMMABLE BASE EDITOR SYSTEMS
#2706ENGINEERED INCOHERENT FEED FORWARD LOOP AND USES THEREOF
#2707METHODS FOR MODIFYING PLASTID GENOMES
#2708CRISPR SYSTEMS IN PLANTS
#2709METHODS FOR CIRCULARIZING LINEAR DOUBLE STRANDED NUCLEIC ACIDS
#2710TARGETING THE PALMOTYLATION/DEPALMOTYLATION CYCLE TO TREAT INFLAMMATORY DISEASES
#2711CHROMATIN REMODELERS TO ENHANCE TARGETED GENE ACTIVATION
#2712Base editing of PCSK9 and methods of using same for treatment of disease
#2713MODIFIED CRISPR RNA AND MODIFIED SINGLE CRISPR RNA AND USES THEREOF
#2714ENZYME COMPOSITIONS AND USES THEREOF
#2715CHEMICALLY MODIFIED GUIDE RNAS FOR GENOME EDITING WITH CAS9
#2716GENE EDITING OF MONOGENIC DISORDERS IN HUMAN HEMATOPOIETIC STEM CELLS -- CORRECTION OF X-LINKED HYPER-IGM SYNDROME (XHIM)
#2717SAFE HARBOR LOCI
#2718METHODS AND COMPOSITIONS FOR IMPROVING PLANT ARCHITECTURE AND YIELD TRAITS
#2719DIRECT REPLACEMENT GENOME EDITING
#2720APPLICATION OF MAL33 GENE DELETION IN IMPROVING TOLERANCE OF SACCHAROMYCES CEREVISIAE TO INHIBITORS IN THE LIGNOCELLULOSE HYDROLYZATES
#2721COMPOSITIONS AND METHODS FOR ENHANCING HOMOLOGOUS RECOMBINATION
#2722Transposase polypeptides and uses thereof
#2723GENOME EDITING USING CAS9 OR CAS9 VARIANT
#2724ZINC FINGER DEGRADATION DOMAINS
#2725METHOD FOR SPECIFICALLY EDITING GENOMIC DNA AND APPLICATION THEREOF
#2726COMPOSITIONS AND METHODS FOR EXPRESSING FACTOR IX FOR HEMOPHILIA B THERAPY
#2727RECOMBINANT HERPESVIRUS OF TURKEYS (HVT) AND PREPARATION METHOD AND USE THEREOF
#2728GENOME ENGINEERING USING CRISPR RNA-GUIDED INTEGRASES
#2729GENOME ENGINEERING METHOD AND GENOME ENGINEERING KIT
#2730Modified excisable MON87701 soybean transgenic insect resistance locus
#2731COMPOSITIONS AND METHODS FOR INHIBITION AND TARGETING OF P97
#2732Kinetically enhanced engineered FnCas9 and its uses thereof
#2733FNCPF1 MUTANT FOR BROAD-SPECTRUM IDENTIFICATION ON PAM SEQUENCE ANS USE THEREOF
#2734POLYPEPTIDE FOR THE THERAPY OF GLOMERULAR KIDNEY DISEASE AND ANALYSIS OF THE COURSE AND PROGNOSIS OF DEPENDENT SYN-DROMES
#2735CELL-PENETRATING PEPTIDE AND USE THEREOF
#2736METHODS OF EDITING A DISEASE-ASSOCIATED GENE USING ADENOSINE DEAMINASE BASE EDITORS, INCLUDING FOR THE TREATMENT OF GENETIC DISEASE
#2737FORMULATIONS
#2738SHUTTLE VECTOR FOR EXPRESSION IN E. COLI AND BACILLI
#2739TAL- effector nuclease (TALEN) -MODIFIED ALLOGENIC CELLS SUITABLE FOR THERAPY
#2740NOVEL MUTATIONS THAT ENHANCE THE DNA CLEAVAGE ACTIVITY OF ACIDAMINOCOCCUS SP. CPF1
#2741METHODS, COMPOSITIONS AND COMPONENTS FOR CRISPR-CAS9 EDITING OF CBLB IN T CELLS FOR IMMUNOTHERAPY
#2742NUCLEASE-MEDIATED PLASMID INTEGRATION
#2743CRISPR-CAS12i systems
#2744Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#2745UBIQUITIN VARIANTS WITH IMPROVED AFFINITY FOR 53BP1
#2746CHEMICALLY MODIFIED GUIDE RNAS FOR GENOME EDITING WITH CAS12B
#2747DETECTION OF GENE LOCI WITH POLYCHROMATIC CRISPR-ASSOCIATED PROTEIN 9
#2748Amino Acid Mediated Gene Delivery and Its Uses
#2749CAS9 mutant genes and polypeptides encoded by same
#2750CELL CLASSIFIER CIRCUITS AND METHODS OF USE THEREOF
#2751DNase H activity of Neisseria meningitidis Cas9
#2752GENOME INTEGRITY ANALYSIS OF VIRUS VECTORS
#2753USE OF EPHB4 AS A TARGET IN SCREENING DRUGS OR MODELS FOR INCREASING INSULIN SENSITIVITY
#2754RNA-guided transcriptional regulation
#2755TARGET-SPECIFIC CRISPR MUTANT
#2756Methods and systems to improve the signal to noise ratio of DNA methylation partitioning assays
#2757NPP1 FUSION PROTEINS
#2758Compositions and methods for treating hemoglobinopathies
#2759HAIRPIN LOOP ENDED SELF-COMPLEMENTARY DOUBLE-STRANDED COVALENTLY CLOSED LINEAR DNA VECTOR, MANUFACTURING SYSTEM AND PROCESS, AND USES OF SAID RESULTING DNA VECTOR
#2760FIELD DEPLOYABLE CRISPR-CAS DIAGNOSTICS AND METHODS OF USE THEREOF
#2761UNIVERSAL DONOR CELLS
#2762STAT3-TARGETED BASE EDITOR THERAPEUTICS FOR THE TREATMENT OF MELANOMA AND OTHER CANCERS
#2763OPTIMIZED CRISPR/CAS9 SYSTEMS AND METHODS FOR GENE EDITING IN STEM CELLS
#2764MODIFIED BACTERIAL RETROELEMENT WITH ENHANCED DNA PRODUCTION
#2765A Method to Produce Targeted Gene Editing Constructs
#2766Guide scaffolds
#2767GENOME EDITING IN SUNFLOWER
#2768RNA-DIRECTED DNA CLEAVAGE BY THE Cas9-crRNA COMPLEX
#2769TRANSCRIPTION MODULATION IN ANIMALS USING CRISPR/CAS SYSTEMS
#2770Organelle genome modification using polynucleotide guided endonuclease
#2771CRISPR/CAS9 SYSTEM FOR MULTISTRAIN HIV-1 TREATMENT
#2772OMNI-59, 61, 67, 76, 79, 80, 81, and 82 CRISPR nucleases
#2773RNA EDITOR-ENHANCED RNA TRANS-SPLICING
#2774INTERNAL STANDARD FOR CRISPR GUIDE RNA
#2775NOVEL CRISPR-CAS SYSTEMS FOR GENOME EDITING
#2776Materials and methods for increasing gene editing frequency
#2777Guide RNA combinations and methods of use
#2778Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#2779COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#2780COMPOSITIONS AND METHODS COMPRISING PLANTS WITH REDUCED LIPOXYGENASE AND/OR DESATURASE ACTIVITIES
#2781Compositions and methods for improved gene editing
#2782NUCLEOBASE EDITORS AND METHODS OF USE THEREOF
#2783NUCLEASE-SCAFFOLD COMPOSITION DELIVERY PLATFORM
#2784Optimized CRISPR-Cas nucleases and base editors and methods of use thereof
#2785ACTIVATION OF LYTIC GENES IN CANCER CELLS
#2786COMPOSITIONS AND METHODS FOR MODULATING FORKHEAD BOX P3 (FOXP3) GENE EXPRESSION
#2787CRISPR-Cas NUCLEASES FROM CPR-ENRICHED METAGENOME
#2788METHODS OF INTRODUCING VARIATION INTO PLANTS AND PRODUCTS PRODUCED THEREFROM
#2789NUCLEASE-MEDIATED MODULATION OF GENE EXPRESSION
#2790COMPOSITIONS AND METHODS FOR MODIFYING A TARGET NUCLEIC ACID
#2791Using proteases to control star activity of restriction enzymes
#2792PSEUDOTYPED RECOMBINANT LYSSAVIRUSES FOR GENE THERAPY
#2793GENETICALLY MODIFIED CLOSTRIDIUM BACTERIA, PREPARATION AND USES OF SAME
#2794GENE EDITING METHODS FOR TREATING SPINAL MUSCULAR ATROPHY
#2795DISSEMINATED NEOPLASIA CELLS AND METHODS OF THEIR USE TO CONTROL INVASIVE OR PEST SPECIES
#2796Inducible CRISPR system expression and applications thereof
#2797PRODRUG INCORPORATED sgRNA SYNTHESIS
#2798Systems and Methods to Identify Genetic Silencers and Applications Thereof
#2799CRISPR-Cas13 crRNA Arrays
#2800OVERLAPPING THERAPEUTIC STRATEGIES FOR CYSTINOSIS TREATMENT AND COSMETIC SKIN DARKENING
#2801COMPOSITIONS AND METHODS FOR TREATING ALPHA-1 ANTITRYPSIN DEFICIENCY
#2802SINGLE NUCLEIC ACID FOR REAL-TIME DETECTION FOR SNP ANALYSIS OF APOE GENE AND DETECTION METHOD USING THE SAME
#2803VITAMIN B6-COUPLED POLYOL-BASED POLYDIXYLITOL GENE TRANSPORTER COMPRISING PEPTIDE BINDING SPECIFICALLY TO CANCER STEM CELL AND CANCER STEM CELL-TARGETED THERAPY TECHNIQUE
#2804Methods of editing DNA methylation
#2805Inhibition of unintended mutations in gene editing
#2806Polypeptides
#2807Guide RNAs with chemical modification for prime editing
#2808COMPOSITIONS AND METHODS FOR IMPROVING HOMOGENEITY OF DNA GENERATED USING A CRISPR/CAS9 CLEAVAGE SYSTEM
#2809GUIDED EXCISION-TRANSPOSITION SYSTEMS
#2810INTRA-GENOMIC HOMOLOGOUS RECOMBINATION
#2811RNA-GUIDED GENOME RECOMBINEERING AT KILOBASE SCALE
#2812Compositions of matter for detection assays
#2813Methods and compositions for prime editing nucleotide sequences
#2814METHODS AND COMPOSITIONS FOR PRODUCTION OF GENETICALLY MODIFIED PRIMARY CELLS
#2815Compositions and Methods for Detecting Molecular Targets on Chromosomal DNA
#2816CELL SPECIFIC, SELF-INACTIVATING GENOMIC EDITING USING CRISPR-CAS SYSTEMS HAVING RNASE AND DNASE ACTIVITY
#2817RECOGNITION SEQUENCES FOR I-CREI-DERIVED MEGANUCLEASES AND USES THEREOF
#2818GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY
#2819ODORLESS CANNABIS PLANT
#2820NOVEL TYPE IV AND TYPE I CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF
#2821Modified excisable DAS68416-4 soybean transgenic herbicide resistance locus
#2822Sequential gene editing in primary immune cells
#2823BASE EDITOR LACKING HNH AND USE THEREOF
#2824NOVEL DESIGN OF GUIDE RNA AND USES THEREOF
#2825SYSTEMS AND METHODS FOR EVALUATING CAS9-INDEPENDENT OFF-TARGET EDITING OF NUCLEIC ACIDS
#2826METHODS FOR LABELING AND TARGETING CELLS
#2827NOVEL CRISPR-CAS SYSTEMS FOR GENOME EDITING
#2828SYSTEMS AND METHODS FOR IN VIVO DUAL RECOMBINASE-MEDIATED CASSETTE EXCHANGE (dRMCE) AND DISEASE MODELS THEREOF
#2829COMPOSITIONS AND METHODS FOR TARGETING, EDITING OR MODIFYING HUMAN GENES
#2830Modified excisable MON87708 soybean transgenic herbicide resistance locus
#2831CRISPR-BASED FOXP3 GENE ENGINEERED T CELLS AND HEMATOPOIETIC STEM CELL PRECURSORS TO TREAT IPEX SYNDROME PATIENTS
#2832COMPOSITIONS AND METHODS FOR USE IN IMMUNOTHERAPY
#2833COMPOSITIONS AND METHODS FOR COMBINATORIAL ASSEMBLY AND SCREENING FOR FUNCTIONAL SITE-DIRECTED NUCLEOTIDE MODIFIERS
#2834MODIFIED IMMUNE CELLS HAVING ADENOSINE DEAMINASE BASE EDITORS FOR MODIFYING A NUCLEOBASE IN A TARGET SEQUENCE
#2835METHODS FOR RAPID CLONING AND EXPRESSION OF HLA CLASS I CELLS
#2836COMPOSITIONS AND METHODS FOR GENOME ENGINEERING
#2837Targeted Translation of RNA with CRISPR-Cas13 to Enhance Protein Synthesis
#2838Modified excisable DAS59122-7 maize transgenic locus
#2839METHODS AND COMPOSITIONS FOR EDITING NUCLEOTIDE SEQUENCES
#2840IN-SERIES SYNTHETIC RECEPTOR AND-GATE CIRCUITS FOR EXPRESSION OF A THERAPEUTIC PAYLOAD BY ENGINEERED CELLS
#2841Modified excisable 5307 maize transgenic locus lacking a selectable marker
#2842Methods and Compositions for Directed Genome Editing
#2843CODON-OPTIMIZED CAS9 ENDONUCLEASE ENCODING POLYNUCLEOTIDE
#2844NOVEL NUCLEOBASE EDITORS AND METHODS OF USING SAME
#2845ENGINEERED CRISPR/CAS13 SYSTEM AND USES THEREOF
#2846CRISPR enzymes and systems
#2847NOVEL PROTOSPACER ADJACENT MOTIF SEQUENCE AND METHOD FOR MODIFYING TARGET NUCLEIC ACID IN GENOME OF CELL BY USING SAME
#2848GENOME EDITING USING CRISPR IN CORYNEBACTERIUM
#2849Recombinant phages comprising transgenes
#2850NOVEL CLASS 2 CRISPR-CAS RNA-GUIDED ENDONUCLEASES
#2851BASIC DOMAIN-DELETED DNASE1-LIKE 3 AND USES THEREOF
#2852THREE-COMPONENT CRISPR/CAS COMPLEX SYSTEM AND USES THEREOF
#2853NUCLEIC ACID SEQUENCE DETECTION BY MEASURING FREE MONORIBONUCLEOTIDES GENERATED BY ENDONUCLEASE COLLATERAL CLEAVAGE ACTIVITY
#2854COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B
#2855COMPOSITIONS FOR SMALL MOLECULE CONTROL OF PRECISE BASE EDITING OF TARGET NUCLEIC ACIDS AND METHODS OF USE THEREOF
#2856METHOD TO ENHANCE GENE EDITING
#2857Effector proteins and methods of use
#2858TRANSPOSON SYSTEMS FOR GENOME EDITING
#2859PREPARATION METHOD FOR DNA NEXT-GENERATION SEQUENCING LIBRARY
#2860ENGINEERED TARGET SPECIFIC NUCLEASES
#2861Methods and compositions for genomic integration
#2862Applications of engineered Cas9 variants on single-base PAM targets
#2863METHODS TO CHARACTERIZE ENZYMES FOR GENOME ENGINEERING
#2864METHODS AND COMPOSITIONS FOR MODIFYING CYTOKININ RECEPTOR HISTIDINE KINASE GENES IN PLANTS
#2865CELLS HAVING HIGH ADAPTABILITY UNDER HYPOXIC CONDITIONS, AND USE THEREOF
#2866GENETICALLY MODIFIED MEGAKARYOCYTE, MODIFIED PLATELET, AND METHODS RESPECTIVELY FOR PRODUCING SAID GENETICALLY MODIFIED MEGAKARYOCYTE AND SAID MODIFIED PLATELET
#2867COMPOSITION FOR SIMULTANEOUSLY MODIFYING AMINO ACIDS OF SITE 736 AND SITE 738 OF PAPN GENE AND APPLICATION THEREOF
#2868COMPOSITIONS AND METHODS FOR TREATING, AMELIORATING, AND/OR PREVENTING DISEASES OR DISORDERS CAUSED BY OR ASSOCIATED WITH DNASE1 AND/OR DNASE1L3 DEFICIENCY
#2869METHOD FOR RECOVERING PHAS FROM A BIOMASS
#2870METHODS, COMPOSITIONS AND COMPONENTS FOR CRISPR-CAS9 EDITING OF TGFBR2 IN T CELLS FOR IMMUNOTHERAPY
#2871B cell receptor modification in B cells
#2872TRANSPOSITION-BASED DIAGNOSTICS METHODS AND DEVICES
#2873TWO-STEP GENE SWAP
#2874GENE EDITING SYSTEMS COMPRISING A NUCLEASE AND USES THEREOF
#2875High Fidelity SpCas9 Nucleases for Genome Modification
#2876SWITCHABLE CAS9 NUCLEASES AND USES THEREOF
#2877CRISPR/CAS SYSTEM AND USES THEREOF
#2878ARC-BASED CAPSIDS AND USES THEREOF
#2879ENGINEERED CRISPR-CAS SYSTEMS AND METHODS FOR SENSITIVE AND SPECIFIC DIAGNOSTICS
#2880CRISPR DNA targeting enzymes and systems
#2881THERAPEUTIC NUCLEASE COMPOSITIONS AND METHODS
#2882CAS9 VARIANTS AND USES THEREOF
#2883CONSTRUCTION OF HIGH-FIDELITY CRISPR/ASCPF1 MUTANT AND USES THEREOF
#2884CRISPR-ASSOCIATED TRANSPOSASE SYSTEMS AND METHODS OF USE THEREOF
#2885METHODS FOR ENGINEERING HIGHLY ACTIVE T CELL FOR IMMUNOTHERAPHY
#2886SYNTHETIC GUIDE RNA, COMPOSITIONS, METHODS, AND USES THEREOF
#2887ENGINEERED IMMUNE KILLER CELL, PREPARATION METHOD THEREFOR AND USE THEREOF
#2888INHIBITION OF DENND5B EXPRESSION FOR TREATING HEPATIC STEATOSIS
#2889METHODS AND COMPOSITIONS FOR MODULATING GENE EXPRESSION
#2890Engineered class 2 type V CRISPR systems
#2891Directed editing of cellular RNA via nuclear delivery of CRISPR/Cas9
#2892PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING ALZHEIMER'S AND USE THEREOF
#2893GENETICALLY ENGINEERED HEMATOPOIETIC STEM CELLS AND USES THEREOF
#2894Polynucleotides encoding engineered meganucleases having specificity for recognition sequences in the dystrophin gene
#2895NUCLEASE CASCADE ASSAY
#2896PROGRAMMABLE ENZYME-ASSISTED SELECTIVE EXPONENTIAL AMPLIFICATION FOR SENSITIVE DETECTION OF RARE MUTANT ALLELES
#2897REGULATABLE EXPRESSION SYSTEMS
#2898GENE EDITING USING A MESSENGER RIBONUCLEIC ACID CONSTRUCT
#2899crRNA:tracrRNA-BASED BINARY LOGIC GATE DESIGN AS A TOOL FOR SYNTHETIC BIOLOGY
#2900Class II, type II CRISPR systems
#2901ENGINEERED FIBROBLASTS AS CELL THERAPY TO TREAT CANCER VIA TUMOR STROMA STABILIZATION
#2902GENOME EDITING USING REVERSE TRANSCRIPTASE ENABLED AND FULLY ACTIVE CRISPR COMPLEXES
#2903IN VITRO AND IN VIVO GENE DELIVERY TO IMMUNE EFFECTOR CELLS USING NANOPARTICLES FUNCTIONALIZED WITH DESIGNED ANKYRIN REPEAT PROTEINS (DARPINS)
#2904A CAS9-PDBD BASE EDITOR PLATFORM WITH IMPROVED TARGETING RANGE AND SPECIFICITY
#2905AFFINITY TAG FOR RECOMBINATION PROTEIN RECRUITMENT
#2906Optimized protein fusions and linkers
#2907COMPOSITIONS AND METHODS OF TREATMENT FOR LYTIC AND LYSOGENIC VIRUSES
#2908CRISPR-ASSOCIATED TRANSPOSON SYSTEMS AND METHODS OF USING SAME
#2909ZINC FINGER NUCLEASE VARIANTS FOR TREATING OR PREVENTING LYSOSOMAL STORAGE DISEASES
#2910System for the biocontrol of white spot syndrome virus (WSSV) in aquaculture
#2911TARGETED INTEGRATION IN MAMMALIAN SEQUENCES ENHANCING GENE EXPRESSION
#2912METHODS FOR MANUFACTURING GENETICALLY ENGINEERED CAR-T CELLS
#2913GENETICALLY CORRECTED CELLS FOR THERAPEUTIC USE
#2914COMPOSITIONS COMPRISING A NUCLEASE AND USES THEREOF
#2915LARGE-SCALE COMBINED CAR TRANSDUCTION AND CRISPR GENE EDITING OF MSC CELLS
#2916Compositions, Methods and Systems for the Delivery of Gene Editing Material to Cells
#2917Compositions and Methods Comprising a TTR Guide RNA and a Polynucleotide Encoding an RNA-Guided DNA Binding Agent
#2918TREATMENT OF CHRONIC PAIN
#2919METHODS FOR TARGETED CELL DEPLETION
#2920CRISPR CASCADE ASSAY
#2921Efficient TCR gene editing in T lymphocytes
#2922CRISPR-CAS10 SYSTEMS AND METHODS FOR PHAGE GENOME EDITING
#2923COMPOSITIONS, METHODS, AND SYSTEMS FOR GENOME EDITING TECHNOLOGY
#2924RETROTRANSPOSONS AND USE THEREOF
#2925ND2006 CAS12A mutant genes and polypeptides encoded by same
#2926CRISPR-based programmable RNA editing
#2927DEVELOPMENT OF DUAL-gRNA APPROACH WITH UNDETECTABLE OFF-TARGET EFFECT TO CORRECT C9ORF72 REPEAT EXPANSION AND C9ORF72 PATHOLOGY
#2928COMPOSITIONS AND METHODS FOR TREATING CEP290-ASSOCIATED DISEASE
#2929METHODS AND COMPOSITIONS FOR KILLING A TARGET BACTERIUM
#2930PROGRAMMABLE DNA NUCLEASE-ASSOCIATED LIGASE AND METHODS OF USE THEREOF
#2931Bioengineered Microbial Spores
#2932Novel Vectors and Uses Thereof
#2933ENGINEERED IMMUNE CELLS WITH REDUCED TOXICITY AND USES THEREOF
#2934ENGINEERING CIRCULAR GUIDE RNAS
#2935Compositions and Methods for TTR Gene Editing and Treating ATTR Amyloidosis Comprising a Corticosteroid or Use Thereof
#2936CULTURES OF AND METHODS OF MANUFACTURING SQUAMOUS CELL CARCINOMA CELLS
#2937GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING LACTATE DEHYDROGENASE A (LDHA) AND USES THEREOF
#2938Treatment Of Cognitive Impairment With Alpha-N-Acetylgalactosaminide Alpha-2,6-Sialyltransferase 5 (ST6GALNAC5) Inhibitors
#2939Methods and products for transfecting cells
#2940COMPOSITIONS AND METHODS FOR THE TARGETING OF RHODOPSIN
#2941USE OF CELLULASE FOR IMPROVEMENT OF SUSTAINABILITY OF DETERGENTS
#2942SYSTEMS AND METHODS FOR LIPID NANOPARTICLE DELIVERY OF GENE EDITING MACHINERY
#2943Modified immune cells having enhanced function and methods for screening for same
#2944COMPOSITIONS AND METHODS FOR THE TARGETING OF HTT
#2945GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING HYDROXYACID OXIDASE 1 (HAO1) AND USES THEREOF
#2946VARIANT CAS9
#2947HSD17B13 VARIANTS AND USES THEREOF
#2948OPTIMIZED ENGINEERED MEGANUCLEASES HAVING SPECIFICITY FOR A RECOGNITION SEQUENCE IN THE HEPATITIS B VIRUS GENOME
#2949SPLIT-ENZYME SYSTEM TO DETECT SPECIFIC DNA IN LIVING CELLS
#2950METHOD FOR DETECTING TARGET NUCLEIC ACID, METHOD FOR DETECTING NUCLEIC ACID-BINDING MOLECULE, AND METHOD FOR EVALUATING NUCLEIC ACID-BINDING ABILITY
#2951DELIVERY, USE AND THERAPEUTIC APPLICATIONS OF THE CRISPR-CAS SYSTEMS AND COMPOSITIONS FOR GENOME EDITING
#2952METHODS AND COMPOSITIONS TO PROMOTING RETINAL REGENERATION USING PROX1 MIGRATION INHIBITOR AS ACTIVE INGREDIENT
#2953Cleaning Compositions comprising Enzymes
#2954DEVICE FOR CONTINUOUSLY PRODUCING AND ANALYZING RNA
#2955CRISPR-CAS EFFECTOR POLYPEPTIDES AND METHODS OF USE THEREOF
#2956Cas9 as a genome engineering platform with novel PAM specificity
#2957Compositions and methods for organ specific delivery of nucleic acids
#2958CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING SICKLE CELL DISEASE
#2959CRISPR/Cas-related methods and compositions for treating Leber's congenital amaurosis 10 (LCA10)
#2960NOVEL TYPE VI CRISPR ENZYMES AND SYSTEMS
#2961SPLIT DEAMINASE BASE EDITORS
#2962METHODS FOR DUAL DNA/PROTEIN TAGGING OF OPEN CHROMATIN
#2963POLYNUCLEOTIDES ENCODING APOA1-RNASE FUSION POLYPEPTIDES
#2964GENE EDITING SYSTEMS COMPRISING A CRISPR NUCLEASE AND USES THEREOF
#2965DELIVERY OF BIOLOGICAL MOLECULES TO PLANT CELLS
#2966REMOVAL OF CONSTRUCTS FROM TRANSFORMED CELLS
#2967METHODS AND COMPOSITIONS INVOLVING CRISPR CLASS 2, TYPE VI GUIDES
#2968COMPOSITIONS AND METHODS FOR EDITING BETA-GLOBIN FOR TREATMENT OF HEMAGLOBINOPATHIES
#2969CAS9 VARIANTS HAVING NON-CANONICAL PAM SPECIFICITIES AND USES THEREOF
#2970MATERIALS AND METHODS FOR ENGINEERING CELLS AND USES THEREOF IN IMMUNO-ONCOLOGY
#2971Engineered CRISPR-Cas9 nucleases with Altered PAM Specificity
#2972CRISPR/CAS-MEDIATED GENE CONVERSION
#2973COMPOSITIONS AND METHODS FOR NON-TOXIC CONDITIONING
#2974NOVEL CRISPR DNA TARGETING ENZYMES AND SYSTEMS
#2975ENGINEERED CELLS WITH IMPROVED PROTECTION FROM NATURAL KILLER CELL KILLING
#2976Lipid-encapsulated dual-cleaving endonuclease for DNA and gene editing
#2977DNASE FUSION POLYPEPTIDES AND RELATED COMPOSITIONS AND METHODS
#2978NUCLEIC ACID PRODUCTS AND METHODS OF ADMINISTRATION THEREOF
#2979Polynucleotides, Compositions, and Methods for Polypeptide Expression
#2980METHOD FOR PROVIDING IMMUNE CELLS WITH ENHANCED FUNCTION
#2981LIGATION-BASED GENE EDITING USING CRISPR NICKASE
#2982Application of CAS protein, method for detecting target nucleic acid molecule and kit
#2983ANTI-BACTERIAL CRISPR COMPOSITIONS AND METHODS
#2984CRISPR/CAS-RELATED METHODS, COMPOSITIONS AND COMPONENTS
#2985Vitro Cleavage of DNA Using Argonaute
#2986DNA modifying enzymes and active fragments and variants thereof and methods of use
#2987BASE-EDITING SYSTEMS
#2988SUPERNEGATIVELY CHARGED PROTEINS AND USES THEREOF
#2989SELECTIVE EXPANSION OF GENE-TARGETED CELLS
#2990CRISPR AND AAV STRATEGIES FOR X-LINKED JUVENILE RETINOSCHISIS THERAPY
#2991RNA GUIDED ERADICATION OF HUMAN JC VIRUS AND OTHER POLYOMAVIRUSES
#2992DUAL SUPRAMOLECULAR NANOPARTICLE VECTORS ENABLE CRISPR/CAS9-MEDIATED KNOCKIN OF RETINOSCHISIN 1 GENE-A POTENTIAL NON-VIRAL THERAPEUTIC SOLUTIONS FOR X-LINKED JUVENILE RETINOSCHISIS
#2993PROGRAMMABLE NUCLEASE COMPOSITIONS AND METHODS OF USE THEREOF
#2994METHODS OF SYNTHESIZING RNA MOLECULES
#2995APPLICATION OF TRANSPORT CARRIER GENE WHICH IMPROVES L-TRYPTOPHAN PRODUCTION EFFICIENCY IN ESCHERICHIA COLI
#2996METHOD OF ENGINEERING HYPOIMMUNOGENIC MUSCLE PRECURSOR CELLS
#2997METHODS AND COMPOSITIONS FOR GENOMIC INTEGRATION
#2998METHOD FOR CONDUCTING SITE-SPECIFIC MODIFICATION ON ENTIRE PLANT VIA GENE TRANSIENT EXPRESSION
#2999ENGINEERED CELLS FOR CONTROLLED PRODUCTION
#3000A CRISPR-CAS9 PLATFORM WITH AN INTRINSIC OFF-SWITCH AND ENHANCED SPECIFICITY