108937 ⎘
Enzymes; Proenzymes; Compositions thereof ; Processes for preparing, activating, inhibiting, separating or purifying enzymes; Hydrolases (3) acting on ester bonds (3.1) Ribonucleases RNAses, DNAses
DNA MODIFYING ENZYMES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#1202Systems targeting PSMA and CA9
#1203CRISPR INDUCED DISRUPTION OF MOGS GENE
#1204CRISPR/CAS9-BASED COMPOSITIONS AND METHODS FOR TREATING RETINAL DEGENERATIONS
#1205COMPOSITIONS AND METHODS FOR INHIBITING THE EXPRESSION OF TMIGD2
#1206DNA modifying enzymes and active fragments and variants thereof and methods of use
#1207CLASS II, TYPE V CRISPR SYSTEMS
#1208COMPOSITIONS AND METHODS FOR SITE-DIRECTED MUTAGENESIS
#1209EPIGENETIC MODULATORS FOR TISSUE REPROGRAMMING
#1210A METHOD FOR IN VIVO GENE THERAPY TO CURE SCD WITHOUT MYELOABLATIVE TOXICITY
#1211COMPOSITIONS AND METHODS FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY (SMA)
#1212MODIFIED ORGANS AND TISSUES
#1213SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#1214SINGLE CELL CHROMATIN IMMUNOPRECIPITATION SEQUENCING ASSAY
#1215REGULATION OF CELLS AND ORGANISMS
#1216METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#1217SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#1218Methods of Treating Rheumatoid Arthritis Using RNA-Guided Genome Editing of HLA Gene
#1219CYTIDINE DEAMINASES AND METHODS OF GENOME EDITING USING THE SAME
#1220MODIFICATION OF BRASSINOSTEROID RECEPTOR GENES TO IMPROVE YIELD TRAITS
#1221COMPOSITIONS AND METHODS COMPRISING PLANTS WITH REDUCED RAFFINOSE FAMILY OLIGOSACCHARIDES AND/OR HIGH PROTEIN CONTENT
#1222METHODS AND COMPOSITIONS FOR REDUCING POLYPHENOL OXIDASE ACTIVITY IN PLANTS
#1223COMPOSITIONS AND METHODS COMPRISING PLANTS WITH MODIFIED SEED PROTEIN AND/OR OIL CONTENT
#1224DOUBLE DECAPITATION OF PLANTS
#1225SYSTEMS AND METHODS FOR AN INTRANASAL DRUG DELIVERY SYSTEM
#1226TARGET SEQUENCE SPECIFIC ALTERATION TECHNOLOGY USING NUCLEOTIDE TARGET RECOGNITION
#1227COMPOSITIONS AND METHODS FOR IMPROVING T CELL PERSISTENCE AND FUNCTION
#1228ADAR SPECIFIC GUIDE RNAS AND USES THEREOF
#1229CRISPR ENZYMES, METHODS, SYSTEMS AND USES THEREOF
#1230FUSION EFFECTOR PROTEINS AND USES THEREOF
#1231ENGINEERED PROTEINS AND METHODS OF USE THEREOF
#1232EFFECTOR PROTEINS AND METHODS OF USE
#1233CHIMERIC PSEUDOTYPED RECOMBINANT RABIES VIRUS
#1234COMPOSITIONS AND METHODS FOR CELLULAR REPROGRAMMING USING CIRCULAR RNA
#1235DELIVERY OF CAS9 VIA ARRDC1-MEDIATED MICROVESICLES (ARMMS)
#1236PROGRAMMABLE NUCLEASE DIAGNOSTIC DEVICE
#1237TREATING DISEASES AND IMPROVING NUCLEIC ACID DELIVERY
#1238MODIFIED IMMUNE CELLS AND METHODS OF USING THE SAME
#1239GENOMIC EDITING OF RBM20 MUTATIONS
#1240CHIMERIC ANTIGEN RECEPTOR TO TARGET TROP-2-POSITIVE CANCERS
#1241LIPID NANOPARTICLE COMPOSITIONS FOR DELIVERY OF MRNA AND LONG NUCLEIC ACIDS
#1242RNASE H2 MUTANTS THAT REDUCE PRIMER DIMERS AND OFF-TARGET AMPLIFICATION IN RHPCR-BASED AMPLICON SEQUENCING WITH HIGH-FIDELITY DNA POLYMERASES
#1243STRATEGIES TO DEVELOP GENOME EDITING SPHERICAL NUCLEIC ACIDS (SNAS)
#1244ENGINEERED NODAVIRAL CARGO DELIVERY SYSTEMS
#1245COMPOSITIONS AND METHODS FOR GENE EDITING
#1246Method for the Generation of Genome Edited Protoplasts from Clonally Propagated Plant Tissue
#1247METHODS AND COMPOSITIONS FOR MODULATING A GENOME
#1248TYPE I-B CRISPR-ASSOCIATED TRANSPOSASE SYSTEMS
#1249NUCLEIC ACID-GUIDED NICKASES
#1250GENE THERAPY FOR THE TREATMENT OF SEVERE COMBINED IMMUNODEFICIENCY (SCID) RELATED TO RAG1
#1251METHOD FOR PRODUCING DIRECTLY REPROGRAMMED NATURAL KILLER CELLS AND USES THEREOF
#1252Cell line for TCR discovery and engineering and methods of use thereof
#1253NUCLEIC ACIDS ENCODING ANCHOR MODIFIED ANTIBODIES AND USES THEREOF
#1254Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism
#1255BICISTRONIC CONSTRUCTS FOR ALLOGENEIC GENE THERAPY
#1256ALTERED EXPRESSION OF Y CHROMOSOME-LINKED ANTIGENS IN HYPOIMMUNOGENIC CELLS
#1257Compositions and Methods for Gene Editing in T Cells Using CRISPR/Cpf1
#1258METHODS FOR GENERATING PRIMARY IMMUNE CELLS
#1259TRANSCRIPTION ACTIVATOR-LIKE EFFECTOR NUCLEASES (TALENS) TARGETING HBV
#1260RARE NUCLEIC ACID DETECTION
#1261BASE EDITING ENZYMES
#1262S. PYOGENES CAS9 MUTANT GENES AND POLYPEPTIDES ENCODED BY SAME
#1263HERBICIDE RESISTANT CANNABIS PLANT
#1264METHODS AND COMPOSITIONS FOR SENSITIZATION OF TUMOR CELLS TO IMMUNE THERAPY
#1265NON-RIBOSOMAL SEQUENCE ENRICHMENT AND SINGLE-STRANDED DNA LIBRARY FOR NUCLEIC ACID GUIDED NUCLEASE TARGETING
#1266TRANS-ACTIVATORS AND METHODS AND USE THEREOF
#1267CLASS II, TYPE II CRISPR SYSTEMS
#1268MODIFIED DOUBLE-STRANDED DONOR TEMPLATES
#1269COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#1270SYSTEMS, METHODS, AND COMPOSITIONS COMPRISING MINIATURE CRISPR NUCLEASES FOR GENE EDITING AND PROGRAMMABLE GENE ACTIVATION AND INHIBITION
#1271Fusion Proteins for CRISPR-based Transcriptional Repression
#1272COMPOSITIONS COMPRISING A VARIANT CAS12I4 POLYPEPTIDE AND USES THEREOF
#1273COMPOSITIONS AND METHODS FOR GENE EDITING
#1274COMPOSITIONS AND METHODS FOR THE TARGETING OF C9orf72
#1275RNA expression modulating or editing method via regulation of Cas13 protein
#1276Yeast Single Nucleotide Polymorphisms for Industrially Relevant Phenotypes
#1277THERAPEUTIC GENE SILENCING WITH CRISPR-CAS13
#1278TRANSDUCTION BUFFER
#1279PROTECTED EFFECTOR CELLS AND USE THEREOF FOR ALLOGENEIC ADOPTIVE CELL THERAPIES
#1280EGFR-TARGETING CHIMERIC ANTIGEN RECEPTOR
#1281CYTOKINE ASSOCIATED TUMOR INFILTRATING LYMPHOCYTES COMPOSITIONS AND METHODS
#1282A METHOD FOR IDENTIFYING PEPTIDE THERAPEUTICS TO TREAT A VARIETY OF CONDITIONS
#1283NUCLEASES FOR SIGNAL AMPLIFICATION
#1284GENE EDITING METHOD FOR INHIBITING ABERRANT SPLICING IN STATHMIN 2 (STMN2) TRANSCRIPT
#1285CAS12I2 FUSION MOLECULES AND USES THEREOF
#1286CRISPR-ASSOCIATED TRANSPOSON SYSTEMS AND METHODS OF USING SAME
#1287GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF CYSTIC FIBROSIS
#1288METHODS AND COMPOSITIONS FOR INSERTION OF ANTIBODY CODING SEQUENCES INTO A SAFE HARBOR LOCUS
#1289MODIFICATION OF BRASSINOSTEROID SIGNALING PATHWAY GENES FOR IMPROVING YIELD TRAITS IN PLANTS
#1290COMPOSITIONS AND METHODS COMPRISING PLANTS WITH INCREASED SEED AMINO ACID CONTENT
#1291MANIPULATED IMMUNOREGULATORY ELEMENT AND IMMUNITY ALTERED THEREBY
#1292GUIDE RNAS FOR CRISPR/CAS EDITING SYSTEMS
#1293METHODS OF MAKING UNBIASED PHAGE LIBRARIES
#1294PROTEIN EXPRESSION
#1295METHODS FOR CONTROLLING MERISTEM SIZE FOR CROP IMPROVEMENT
#1296SYSTEMS AND METHODS FOR CAPTURE OF CIRCULATING FREE DNA
#1297METHOD FOR DIGESTING NUCLEIC ACID IN A SAMPLE
#1298DNA MODIFYING ENZYMES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#1299EFFECTOR PROTEINS AND USES THEREOF
#1300ESTIMATION OF PHENOTYPES USING LARGE-EFFECT EXPRESSION VARIANTS
#1301Polynucleotides, Compositions, and Methods for Genome Editing
#1302CLASS 2 CRISPR/CAS COMPOSITIONS AND METHODS OF USE
#1303CIITA TARGETING ZINC FINGER NUCLEASES
#1304SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#1305FANZORS ARE RNA-GUIDED NUCLEASES ENCODED IN EUKARYOTIC GENOMES
#1306TREATMENT FOR HSV-1 USING A MEGANUCLEASE
#1307CRISPR-ASSOCIATED TRANSPOSON SYSTEMS AND METHODS OF USING SAME
#1308POLYPEPTIDE VARIANTS
#1309METHODS OF TREATING MITOCHONDRIAL DISORDERS
#1310INHIBITORS OF DNA-DEPENDENT PROTEIN KINASE AND COMPOSITIONS AND USES THEREOF
#1311NOVEL AAV SEROTYPES DERIVED FROM A LIBRARY SCREEN
#1312ENGINEERED MEGANUCLEASES HAVING SPECIFICITY FOR A RECOGNITION SEQUENCE IN THE HYDROXYACID OXIDASE 1 GENE
#1313Modified Guide RNAs for Gene Editing
#1314GENE EDITING TO IMPROVE JOINT FUNCTION
#1315GENE THERAPY FOR THE TREATMENT OF HYPER-IgE SYNDROME (HIES) BY TARGETED GENE INTEGRATION
#1316TRANSGENIC ANIMALS AND TRANSGENIC EMBRYOS PRODUCING AN ENGINEERED NUCLEASE
#1317CELL-BASED ASSAY FOR QUANTIFYING THE POTENCY AND EFFICACY OF CANNABINOIDS AND/OR TERPENOIDS, AND METHODS OF USE THEREOF
#1318ENDONUCLEASE SYSTEMS
#1319RNA-guided nucleases and active fragments and variants thereof and methods of use
#1320TARGETED DEAMINASE AND BASE EDITING USING SAME
#1321RNA-Guided Human Genome Engineering
#1322METHODS AND COMPOSITIONS FOR MODIFYING SHADE AVOIDANCE IN PLANTS
#1323METHODS AND COMPOSITIONS FOR MODIFYING SHADE AVOIDANCE IN PLANTS
#1324Organelle genome modification using polynucleotide guided endonuclease
#1325COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B VIRUS INFECTION
#1326METHODS AND COMPOSITIONS USING ONE-SIDED TRANSPOSITION
#1327SYSTEMS, METHODS, AND COMPOSITIONS FOR RNA-GUIDED RNA-TARGETING CRISPR EFFECTORS
#1328DNASE FUSION POLYPEPTIDES AND RELATED COMPOSITIONS AND METHODS
#1329ENGINEERED NATURAL KILLER (NK) CELLS AND COMPOSITIONS AND METHODS THEREOF
#1330METHODS OF TREATING MITOCHONDRIAL DISORDERS
#1331ENGINEERED CELLS FOR THERAPY
#1332SYSTEMS AND METHODS FOR PRODUCING PROGENY WITH SELECTIVE TRAITS
#1333METHODS FOR IMPROVING RESISTANCE TO SOYBEAN RUST
#1334METHODS AND SYSTEMS FOR IDENTIFYING TARGET GENES
#1335COMPOSITIONS AND METHODS FOR LARGE-SCALE IN VIVO GENETIC SCREENING
#1336An Isothermal Diagnostic Test that Utilizes a Cas Protein and a Polymerase
#1337METHOD FOR MODIFYING TARGET SITE IN GENOME OF EUKARYOTIC CELL, AND METHOD FOR DETECTING PRESENCE OR ABSENCE OF NUCLEIC ACID SEQUENCE TO BE DETECTED AT TARGET SITE
#1338NOVEL PROCESSES FOR THE PRODUCTION OF OLIGONUCLEOTIDES
#1339GENETIC MODIFICATION
#1340GLOBIN GENE THERAPY FOR TREATING HEMOGLOBINOPATHIES
#1341METHODS AND COMPOSITIONS FOR MODIFYING SHADE AVOIDANCE IN PLANTS
#1342DELAY OR PREVENTION OF BROWNING IN BANANA FRUIT
#1343LIBRARY CONSTRUCTION METHOD BASED ON LONG OVERHANG SEQUENCE LIGATION
#1344Tools and Methods for Mycoplasma Engineering
#1345BIFUNCTIONAL CHEMICAL EPIGENENTIC MODIFIERS AND METHODS OF USE
#1346IMPROVED CYTOSINE TO GUANINE BASE EDITORS
#1347IMPROVED CAS 12A/NLS MEDIATED THERAPEUTIC GENE EDITING PLATFORMS
#1348SYSTEMS, COMPOSITIONS, AND METHODS INVOLVING RETROTRANSPOSONS AND FUNCTIONAL FRAGMENTS THEREOF
#1349ENGRAFTABLE CELL-BASED IMMUNOTHERAPY FOR LONG-TERM DELIVERY OF THERAPEUTIC PROTEINS
#1350METHODS AND MATERIALS FOR TREATING MUSCULAR DYSTROPHY
#1351COMPOSITIONS AND METHODS TO PROGRAM THERAPEUTIC CELLS USING TARGETED NUCLEIC ACID NANOCARRIER
#1352GENETICALLY MODIFIED NK CELLS AND USES THEREOF
#1353METHOD FOR CONTROLLING SLIME IN A PULP OR PAPER MAKING PROCESS
#1354MULTI COLOR WHOLE-GENOME MAPPING AND SEQUENCING IN NANOCHANNEL FOR GENETIC ANALYSIS
#1355CRISPR-CAS12A REACTION FOR RAPID AND HIGHLY SENSITIVE ISOTHERMAL NUCLEIC ACID DETECTION
#1356PEPTIDE NUCLEIC ACIDS FOR SPATIOTEMPORAL CONTROL OF CRISPR-CAS BINDING
#1357CYTOSOLIC DELIVERY OF GENOME EDITING TOOLS
#1358VECTOR-FREE DELIVERY OF GENE EDITING PROTEINS AND COMPOSITIONS TO CELLS AND TISSUES
#1359RNA-Guided Human Genome Engineering
#1360METHODS AND COMPOSITIONS FOR MODIFYING SHADE AVOIDANCE IN PLANTS
#1361GRAFTED PLANT FOR DELIVERY OF GENOME EDITING REAGENTS
#1362NUCLEIC ACID NANOPARTICLES, PHARMACEUTICAL COMPOSITIONS, AND METHODS OF USE THEREOF
#1363GENE EDITING FOR EXPRESSION OF FUNCTIONAL FACTOR VIII FOR THE TREATMENT OF HEMOPHILIA
#1364METHODS FOR CONTROLLING MERISTEM SIZE FOR CROP IMPROVEMENT
#1365ISOLATED CAS13 PROTEIN AND USE THEREOF
#1366CRISPR-TRANSPOSON SYSTEMS FOR DNA MODIFICATION
#1367CRISPR/CAS9-BASED REPRESSORS FOR SILENCING GENE TARGETS IN VIVO AND METHODS OF USE
#1368Compositions and methods for making epigenetic modifications
#1369TCRS SPECIFIC FOR MINOR HISTOCOMPATIBILITY (H) ANTIGEN HA-1 AND USES THEREOF
#1370POLYOXYETHYLENE DERIVATIVES AND CONJUGATES THEREOF
#1371HYPOIMMUNE CELLS
#1372SGRNA AND CONSTRUCTING DUAL PIG MODEL OF SEVERE IMMUNODEFICIENCY AND LIVER INJURY AND USE THEREOF
#1373METHODS OF TREATMENT WITH AMINOLEVULINIC ACID SYNTHASE 2 (ALAS2) MODULATORS
#1374DIMERIZATION SCREENING ASSAYS
#1375SYNTHETIC GENOMIC SAFE HARBORS AND METHODS THEREOF
#1376ENGINEERED GUIDE RNA SCAFFOLDS AND METHODS THEROF FOR ENHANCED GENOME EDITING
#1377RNA POLYMERASE III PROMOTERS AND METHODS OF USE
#1378RNA-GUIDED CAS NUCLEASES AND USES THEREOF IN DIAGNOSTICS AND THERAPY
#1379RNA GUIDED ERADICATION OF HERPES SIMPLEX TYPE I AND OTHER RELATED HUMAN HERPESVIRUSES
#1380METHODS OF ENHANCING AND EXPEDITING EXPRESSION OF ANTIBODIES
#1381SUPPRESSION OF PAIN BY GENE EDITING
#1382EFFECTOR PROTEINS AND METHODS OF USE
#1383CAS9 NICKASE-MEDIATED GENE EDITING
#1384ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE HEPATITIS B VIRUS GENOME
#1385ENGINEERED PROTEINS AND METHODS OF USE THEREOF
#1386VECTOR MANUFACTURING PROCESSES
#1387CRISPR-Cas9 Knock-out of SHP-1/2 to Reduce T cell Exhaustion in Adoptive Cell Therapy
#1388Compositions and methods for enhancing adoptive T cell therapeutics
#1389METHOD FOR PURIFYING A CATIONIC PROTEIN FRACTION AND FRACTION THUS OBTAINED
#1390ADENO-ASSOCIATED VIRUS VIRIONS AND METHODS OF USE THEREOF
#1391PD-1 GENE-EDITED TUMOR INFILTRATING LYMPHOCYTES AND USES OF SAME IN IMMUNOTHERAPY
#1392Subject-Specific Tumor Inhibiting Cells and the Use Thereof
#1393CRYOGENICALLY ARRAYABLE STABLE TRANSFECTION
#1394CRISPR-Cas13 System, Kit and Method for Detecting SARS-CoV-2
#1395Lipid Compositions and Methods for Delivery to Immune Cells
#1396CRISPR TRANSIENT EXPRESSION CONSTRUCT (CTEC)
#1397ADVANCED GENOME EDITING
#1398AUTOMATED CELL PROCESSING METHODS, MODULES, INSTRUMENTS, AND SYSTEMS
#1399GENE EDITING IN PRIMARY IMMUNE CELLS USING CELL PENETRATING CRISPR-CAS SYSTEM
#1400DUPLEX-SPECIFIC DNASES
#1401USE OF A FUSION PROTEIN FOR INDUCING GENETIC MODIFICATIONS BY TARGETED MEIOTIC RECOMBINATION
#1402COMPOSITIONS, METHODS AND USES FOR TREATING CYSTIC FIBROSIS AND RELATED DISORDERS
#1403GENE EDITING THERAPY FOR HIV INFECTION VIA DUAL TARGETING OF HIV GENOME AND CCR5
#1404GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING TRANSTHYRETIN (TTR) AND USES THEREOF
#1405NOVEL TARGETS FOR ENHANCING ANTI-TUMOR IMMUNITY
#1406CHIMERIC TRANSGENIC IMMUNOGLOBULIN MICE WITH AN ALTERED HEAVY CHAIN LOCUS AND METHODS OF MAKING AND USING SAME
#1407PAIRED-CELL PROFILING SYSTEMS FOR HIGH-THROUGHPUT SCREENING SYNCYTIUM FORMATION
#1408SYSTEMS AND METHODS FOR REGULATING TARGET GENES
#1409Degenerate CRISPR Cas13a crRNAs for Detection of Highly Variable RNA Sequences
#1410COMPLEX FOR GENOME EDITING HAVING STABILITY AND FEW SIDE-EFFECTS, AND NUCLEIC ACID CODING SAME
#1411VIRAL VECTOR PRODUCTION SYSTEMS, ENGINEERED CELLS FOR VIRAL VECTOR PRODUCTION, AND METHODS OF USE THEREOF
#1412PRODUCTS AND METHODS FOR TREATMENT OF DYSTROPHIN-BASED MYOPATHIES USING CRISPR-CAS9 TO CORRECT DMD EXON DUPLICATIONS
#1413Multi-Genome Editor Construct and Uses Thereof
#1414ENGINEERED CELLS FOR PRODUCING OF THERAPEUTIC AGENTS TO BE DELIVERED BY A HYBRID BIOELECTRONIC DEVICE
#1415DMP PROTEIN, ENCODING GENE AND USE THEREOF
#1416PHAGE-DERIVED PARTICLES FOR IN SITU DELIVERY OF DNA PAYLOAD INTO C. ACNES POPULATION
#1417GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING HYDROXYACID OXIDASE 1 (HAO1) AND USES THEREOF
#1418COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF FRATAXIN (FXN)
#1419ENGINEERED GUIDE RNA FOR OPTIMIZED CRISPR/CAS12F1 SYSTEM AND USE THEREOF
#1420COMPOSITIONS AND METHODS OF MODIFYING A PLANT GENOME TO PRODUCE A MS9, MS22, MS26, OR MS45 MALE-STERILE PLANT
#1421Nucleic acid molecules encoding DNA modifying enzymes and active fragments and variants thereof and compositions comprising the same
#1422ENGINEERED CLASS 2, TYPE V REPRESSOR SYSTEMS
#1423HEAT-RESISTANT ENDONUCLEASE AND GENE EDITING SYSTEM MEDIATED BY HEAT-RESISTANT ENDONUCLEASE
#1424CLEAVAGE-INACTIVE CAS12F1, CLEAVAGE-INACTIVE CAS12F1-BASED FUSION PROTEIN, CRISPR GENE-EDITING SYSTEM COMPRISING SAME, AND PREPARATION METHOD AND USE THEREOF
#1425ENGINEERED STABLE NUCLEIC ACID-GUIDED NUCLEASES
#1426COMPOSITIONS AND METHODS FOR MODULATING SECRETED FRIZZLED RECEPTOR PROTEIN 1 (SFRP1) GENE EXPRESSION
#1427TRANSCRIPTION ACTIVATOR-LIKE EFFECTOR (TALE) - LYSINE-SPECIFIC DEMETHYLASE 1 (LSD1) FUSION PROTEINS
#1428ENGINEERED CELLS FOR THERAPY
#1429MODIFIED MAMMALIAN CELLS
#1430GENE THERAPY FOR WET AGE-RELATED MACULAR DEGENERATION USING IPSC-DERIVED CELLS AS VECTORS
#1431COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF METHYL-CPG BINDING PROTEIN 2 (MECP2)
#1432Precise Excisions of Portions of Exon 51 for Treatment of Duchenne Muscular Dystrophy
#1433HBB-MODULATING COMPOSITIONS AND METHODS
#1434SYNTHETIC EXOSOMES (SE) FOR CNS DELIVERY OF CRISPR FOR GENE EDITING IN BRAIN DISORDERS
#1435GENETIC MODIFICATION OF HEPATOCYTES
#1436COMPOSITIONS AND METHODS TO TRANSFECT, TEST, AND TREAT SKIN CELLS
#1437CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR IMPROVING TRANSPLANTATION
#1438Detection of nucleic acid and non-nucleic acid target molecules
#1439GENOME EDITING METHOD
#1440METHODS FOR IMPROVED HOMOLOGOUS RECOMBINATION AND COMPOSITIONS THEREOF
#1441METHODS FOR DELIVERING GENOME EDITING MOLECULES TO THE NUCLEUS OR CYTOSOL OF A CELL AND USES THEREOF
#1442COMPOSITIONS AND METHODS FOR ADENO-ASSOCIATED VIRAL PRODUCTION
#1443CRISPR/CAS SYSTEM AND METHOD FOR GENOME EDITING AND MODULATING TRANSCRIPTION
#1444miRNA Switches for RNA-Triggered Control of RNA Interference
#1445SYSTEM AND METHODS FOR INSERTION AND EDITING OF LARGE NUCLEIC ACID FRAGMENTS
#1446GENE ASSEMBLY FROM OLIGONUCLEOTIDE POOLS
#1447METHODS FOR MODULATING CAS-EFFECTOR ACTIVITY
#1448METHODS AND COMPOSITIONS FOR MODULATING A GENOME
#1449URACIL STABILIZING PROTEINS AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#14507-Morpholino-L,6-Naphthyridin-5-yl Derivatives and Pharmaceutical Compositions Thereof Useful as DNA-PK Inhibitor
#1451METHODS FOR STRATIFYING SUBJECTS FOR FETAL HEMOGLOBIN REINDUCTION
#1452COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#1453ENZYME-PORE CONSTRUCTS
#1454Sample splitting for multiplexed detection of nucleic acids without amplification
#1455COMPOSITIONS AND METHODS FOR INCREASING EFFICIENCY OF PRECISE EDITING REPAIR
#1456Increasing Specificity for RNA-Guided Genome Editing
#1457Cas9/RNA Complexes for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#1458HOST FACTORS THAT ENHANCE VIRAL PRODUCTION VIA VIRALLY DRIVEN FITNESS-BASED CRISPR SCREENING
#1459DNase I Variants, Compositions, Methods, and Kits
#1460SYNTHETIC CAS PROTEINS
#1461NON-VIRAL HOMOLOGY MEDIATED END JOINING
#1462COMBINED TRANSPOSON-MEDIATED INTEGRATION AND TARGETED INTEGRATION OF NUCLEIC ACIDS INTO HOST CELLS
#1463HUMAN IMMUNOGLOBULIN HEAVY CHAIN LONG CDR3 TRANSGENE CONSTRUCTS AND USES THEREOF
#14647-Morpholino-1,6-Naphthyridin-5-yl Derivatives and Pharmaceutical Compositions Thereof Useful as DNA-PK Inhibitor
#1465COMPOSITION FOR PREVENTING OR TREATING PROGERIA AND NATURAL AGING THROUGH GENE EDITING
#1466CD-90 Targeted Lipid Nanoparticles
#1467COMPOSITIONS AND METHODS FOR TREATING ACUTE MYELOID LEUKEMIA
#1468TREATMENT OF RETINITIS PIGMENTOSA USING ENGINEERED MEGANUCLEASES
#1469COMPOSITIONS AND METHODS FOR CD123 MODIFICATION
#1470COMPOSITIONS COMPRISING NULLOMERS AND METHODS OF USING THE SAME FOR CANCER DETECTION AND DIAGNOSIS
#1471METHODS FOR ANALYZING NUCLEIC ACID SEQUENCES
#1472METHODS AND COMPOSITIONS FOR SEQUENCING LIBRARY NORMALIZATION
#1473RECOMBINANT CELL AND METHOD FOR PRODUCING ENDOGENOUS POLYPEPTIDE
#1474CRISPR-CAS3 SYSTEMS FOR TARGETED GENOME ENGINEERING
#1475CONTROLLED GENE EXPRESSION METHODS AND MEANS
#1476ENGINEERED TARGET SPECIFIC NUCLEASES
#1477MATERIALS AND METHODS FOR TREATMENT OF GLYCOGEN STORAGE DISEASE TYPE 1A
#1478METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#1479HOMOLOGOUS RECOMBINATION VIA TRANSCRIPTIONAL ACTIVATION
#1480EXPRESSION VECTORS, BACTERIAL SEQUENCE-FREE VECTORS, AND METHODS OF MAKING AND USING THE SAME
#1481MODIFIED ORTHOPOXVIRUS VECTORS
#1482TRANSGENIC CORN EVENT ZM_CSM63715 AND METHODS FOR DETECTION AND USES THEREOF
#1483TOXIN-FREE ALOE AND METHODS OF MAKING SAME
#1484QPT GENE ENGINEERED PLANT CELL AND USING METHOD OF THE SAME
#1485CHLOROPLAST CYTOSINE BASE EDITORS AND MITOCHONDRIA CYTOSINE BASE EDITORS IN PLANTS
#1486SEMI-RATIONAL GENOME EVOLUTION ENGINEERING METHOD FOR PLANTS
#1487COMPOSITIONS FOR GENOME EDITING
#1488RNA-TRIGGERED PROTEIN CLEAVAGE AND APPLICATIONS BY THE CRISPR CAS7-11-CSX29 COMPLEX
#1489TRANSCRIPTIONAL PROGRAMMING IN A BACTEROIDES CONSORTIUM
#1490SITE-SPECIFIC GENOME MODIFICATION TECHNOLOGY
#1491MODIFIED NUCLEIC ACIDS, HYBRID GUIDE RNAS, AND USES THEREOF
#1492TUNING CRISPR/CAS9 ACTIVITY WITH CHEMICALLY MODIFIED NUCLEOTIDE SUBSTITUTIONS
#1493DNASE 1-LIKE 2 ENGINEERED FOR MANUFACTURING AND USE IN THERAPY
#1494RATIONALLY-DESIGNED MEGANUCLEASES WITH ALTERED SEQUENCE SPECIFICITY AND DNA-BINDING AFFINITY
#1495Engineered nucleic acid-guided nucleases
#1496FUSION MOLECULES OF RATIONALLY-DESIGNED DNA-BINDING PROTEINS AND EFFECTOR DOMAINS
#1497METHODS AND COMPOSITIONS FOR IN VIVO GENE EDITING BASED CELL-TYPE-SPECIFIC CELLULAR ENGINEERING
#1498COMPOSITIONS AND METHODS FOR EFFICIENT GENOME EDITING
#1499METHODS FOR EXPANDING REGULATORY T CELLS
#1500Programmed Cell Death Protein 1 (PD1) Compositions and Methods for Cell-Based Therapy