114469 ⎘
Oxidoreductases acting on paired donors, with incorporation or reduction of molecular oxygen (1.14) with reduced pteridine as one donor, and incorporation of one atom of oxygen (1.14.16) Phenylalanine 4-monooxygenase (1.14.16.1)
AAV PIGGYBAC TRANSPOSON POLYNUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREFOR
#2TARGETED INTEGRATION AT ALPHA-GLOBIN LOCUS IN HUMAN HEMATOPOIETIC STEM AND PROGENITOR CELLS
#3COMPOSITIONS AND METHODS FOR THE MANAGEMENT AND TREATMENT OF PHENYLKETONURIA
#4Biosynthesis of Phenylpropanoid Compounds
#5HUMAN PAH EXPRESSION CASSETTE FOR TREATMENT OF PKU BY LIVER-DIRECTED GENE REPLACEMENT THERAPY
#6ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR RESTORING PAH GENE FUNCTION AND METHODS OF USE THEREOF
#7STABLE EXPRESSION OF AAV VECTORS IN JUVENILE SUBJECTS
#8LIPID NANOPARTICLES CONTAINING POLYNUCLEOTIDES ENCODING PHENYLALANINE HYDROXYLASE AND USES THEREOF
#9COMPOSITIONS AND METHODS FOR TREATING PHENYLKETONURIA
#10Auxotrophic Cells for Virus Production and Compositions and Methods of Making
#11Process of Preparing mRNA-Loaded Lipid Nanoparticles
#12CLOSED-ENDED DNA VECTORS AND USES THEREOF FOR EXPRESSING PHENYLALANINE HYDROXYLASE (PAH)
#13ADIPOGENIC CELL COMPOSITIONS AND METHODS
#14METHODS AND COMPOSITIONS FOR EXPRESSING PHENYLALANINE HYDROXYLASE
#15PHENYLALANINE HYDROXYLASE VARIANTS AND USES THEREOF
#16ENGINEERED BACTERIAL STRAINS COMPRISING A TRANSGENE
#17ADENO ASSOCIATED VIRUS BASED GENE THERAPY FOR PHENYLKETONURIA
#18MRNA THERAPY FOR PHENYLKETONURIA
#19ADENO-ASSOCIATED VIRUS PACKAGING SYSTEMS
#20NON-VIRAL DNA VECTORS AND USES THEREOF FOR EXPRESSING PHENYLALANINE HYDROXYLASE (PAH) THERAPEUTICS
#21METHODS OF CELL SELECTION
#22GENE THERAPY FOR TREATING PHENYLKETONURIA
#23OPTIMIZED PHENYLANANINE HYDROXYLASE EXPRESSION
#24GENE THERAPY METHODS
#25Human PAH expression cassette for treatment of PKU by liver-directed gene replacement therapy
#26MULTIMERIC CODING NUCLEIC ACID AND USES THEREOF
#27PHARMABIOTIC TREATMENTS FOR METABOLIC DISORDERS
#28Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof
#29GENERATION OF IMPROVED HUMAN PAH FOR TREATMENT OF SEVERE PKU BY LIVER-DIRECTED GENE REPLACEMENT THERAPY
#30Methods of treating phenylketonuria
#31VECTORS AND METHODS OF USE
#32Optimized microbial cells for production of melatonin and other compounds
#33Polynucleotides encoding phenylalanine hydroxylase for the treatment of phenylketonuria
#34VECTORS WITH PROMOTER AND ENHANCER COMBINATIONS FOR TREATING PHENYLKETONURIA
#35VECTORS AND METHODS OF USE
#36Multimeric coding nucleic acid and uses thereof
#37Compositions and methods for treating phenylketonuria
#38Compositions and methods for treating phenylketonuria
#39METHODS OF ATTACHING A MOLECULE-OF-INTEREST TO A MICROTUBE
#40METHOD OF ATTACHING A CELL-OF-INTEREST TO A MICROTUBE
#41STABLE EXPRESSION OF AAV VECTORS IN JUVENILE SUBJECTS
#42TYROSINE PROTOTROPHY
#43Gene therapy for treating Phenylketonuria
#44Multimeric coding nucleic acid and uses thereof
#45mRNA therapy for phenylketonuria
#46Optimized microbial cells for production of melatonin and other compounds
#47Microbial approach for the production of 5-hydroxytryptophan
#48Process of Preparing mRNA-Loaded Lipid Nanoparticles
#49Allosteric activators for treatment of phenylketonuria
#50Messenger UNA molecules and uses thereof
#51Multimeric coding nucleic acid and uses thereof
#52Microbial approach for the production of 5-hydroxytryptophan
#53MRNA therapy for phenylketonuria
#54METHODS OF ATTACHING A MOLECULE-OF-INTEREST TO A MICROTUBE
#55Methods of expressing products in mammalian cells
#56Compositions, methods, and devices for dialysis
#57MESSENGER UNA MOLECULES AND USES THEREOF
#58COMPOSITION OF ERYTHROCYTES ENCAPSULATING PHENYLALANINE HYDROXYLASE AND THERAPEUTIC USE THEREOF
#59MRNA therapy for phenylketonuria
#60METHOD OF MODULATING PHENYLALANINE HYDROXYLASE STRUCTURE AND FUNCTION
#61Selectable markers and related methods
#62Methods and compositions for treating phenylketonuria
#63Methods of attaching a molecule-of-interest to a microtube
#64Method of attaching a cell-of-interest to a microtube
#65Use of electrospun microtubes for drug delivery
#66Compositions and methods relating to reduction of symptoms of autism
#67Methods of treating amino acid metabolic disorders using recombinant adeno-associated virus virions