114921 ⎘
Transferases transferring one-carbon groups (2.1); Carboxy- and carbamoyltransferases (2.1.3) Ornithine carbamoyltransferase (2.1.3.3)
COMPOSITIONS AND METHODS FOR TREATING ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#2METHODS FOR PURIFICATION OF MESSENGER RNA
#3ADENO-ASSOCIATED VIRUS VIRION FOR TREATING ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#4MICROORGANISM WITH L-ORNITHINE PRODUCTION CAPABILITY AND METHOD FOR PRODUCING L-ORNITHINE USING SAME
#5COMPOSITIONS AND METHODS FOR FACILITATING DELIVERY OF SYNTHETIC NUCLEIC ACIDS TO CELLS
#6IMPROVED BIOTECHNOLOGICAL METHOD FOR PRODUCING GUANIDINO ACETIC ACID (GAA) BY INACTIVATION OF AN AMINO ACID EXPORTER
#7L-AMINO ACID-PRODUCING MICROORGANISM HAVING WEAKENED CARBAMOYL PHOSPHATE SYNTHASE ACTIVITY, AND L-AMINO ACID PRODUCTION METHOD USING SAME
#8METHOD FOR THE FERMENTATIVE PRODUCTION OF GUANIDINOACETIC ACID
#9IMPROVED BIOTECHNOLOGICAL METHOD FOR PRODUCING GUANIDINO ACETIC ACID (GAA) BY USING NADH-DEPENDENT DEHYDROGENASES
#10COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#11Lyophilized Pharmaceutical Compositions Comprising A Lipid Nanoparticle
#12COMPOSITION AND METHODS FOR TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#13COMPOSITIONS AND METHODS FOR THE TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#14Lyophilized Pharmaceutical Compositions Comprising a Lipid Nanoparticle
#15CATIONIC POLYMERS
#16COMPOSITION AND METHODS INCLUDING RECOMBINANT VIRUSES MODULATING ARGININE BIOSYNTHESIS
#17POLYNUCLEOTIDES ENCODING ORNITHINE TRANSCARBAMYLASE FOR THE TREATMENT OF UREA CYCLE DISORDERS
#18LIPID NANOPARTICLES AND POLYNUCLEOTIDES ENCODING ORNITHINE TRANSCARBAMYLASE FOR THE TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#19COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#20Process of Preparing mRNA-Loaded Lipid Nanoparticles
#21COMPOSITIONS AND METHODS FOR TREATING ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#22COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#23COMPOSITIONS USEFUL IN TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#24COMPOSITIONS AND METHODS FOR THE TREATMENT OF METABOLIC LIVER DISORDERS
#25SUBCUTANEOUS DELIVERY OF MESSENGER RNA
#26ORNITHINE TRANSCARBAMYLASE (OTC) CONSTRUCTS AND METHODS OF USING THE SAME
#27Cleavable lipids
#28MULTIMERIC CODING NUCLEIC ACID AND USES THEREOF
#29Composition and methods for treatment of ornithine transcarbamylase deficiency
#30mRNA FOR USE IN TREATMENT OF HUMAN GENETIC DISEASES
#31Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#32COMPOSITIONS AND METHODS FOR THE TREATMENT OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY
#33Arginine supplementation to improve efficiency in gas fermenting acetogens
#34Messenger RNA therapy for the treatment of ornithine transcarbamylase deficiency
#35Methods For Purification of Messenger RNA
#36Methods for purification of messenger RNA
#37Cationic polymers
#38Microorganism for producing ornithine and process for producing ornithine using them
#39Compositions and methods for facilitating delivery of synthetic nucleic acids to cells
#40Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#41FUSION PROTEINS
#42Ornithine transcarbamylase coding polyribonucleotides and formulations thereof
#43Polynucleotides encoding ornithine transcarbamylase for the treatment of urea cycle disorders
#44Cleavable lipids
#45Microorganisms for producing putrescine or ornithine and process for producing putrescine or ornithine using them
#46Compositions and methods for treating ornithine transcarbamylase deficiency
#47Multimeric coding nucleic acid and uses thereof
#48Stable gene transfer to proliferating cells
#49Polynucleotides and vectors for the expression of transgenes
#50Cleavable lipids
#51Subcutaneous delivery of messenger RNA
#52Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#53Multimeric coding nucleic acid and uses thereof
#54Composition and methods for treatment of ornithine transcarbamylase deficiency
#55Microorganisms having putrescine productivity and process for producing putrescine using the same
#56Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#57Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#58Methods for purification of messenger RNA
#59Methods for purification of messenger RNA
#60MRNA for use in treatment of human genetic diseases
#61Microorganisms for producing putrescine or ornithine and process for producing putrescine or ornithine using them
#62Cleavable lipids
#63Process of Preparing mRNA-Loaded Lipid Nanoparticles
#64Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#65L-ornithine production in eukaryotic cells
#66Disease model pig exhibiting stable phenotype, and production method thereof
#67Messenger UNA molecules and uses thereof
#68Messenger RNA therapy for the treatment of ornithine transcarbamylase deficiency
#69Cleavable Lipids
#70Multimeric coding nucleic acid and uses thereof
#71Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#72Stable Gene Transfer to Proliferating Cells
#73Arginine supplementation to improve efficiency in gas fermenting acetogens
#74Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#75Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#76Compositions useful in treatment of ornithine transcarbamylase (OTC) deficiency
#77Microorganisms having putrescine productivity and process for producing putrescine using the same
#78Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#79MESSENGER UNA MOLECULES AND USES THEREOF
#80mRNA for use in treatment of human genetic diseases
#81Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#82Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#83mRNA for use in treatment of human genetic diseases
#84Cleavable lipids
#85Microorganisms for producing putrescine and method for producing putrescine using same
#86Microorganisms having improved ornithine-producing ability and method for producing ornithine using the same
#87mRNA for use in treatment of human genetic diseases
#88Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#89Adeno-associated virus (AAV) serotype 8 sequences, vectors containing same, and uses therefor
#90Adeno-associated virus (AAV) serotype 8 sequences, vectors containing the same, and uses therefor