116231 ⎘
Hydrolases acting on ester bonds (3.1); Carboxylic ester hydrolases (3.1.1) Retinoid isomerohydrolase (3.1.1.64)
RELATIVE POTENCY ASSAY FOR VIRAL VECTOR ENCODING ISOMEROHYDROLASES
#2A SYSTEM FOR AN OCULAR GENE THERAPY AND A PROCESS FOR PREPARING THEREOF
#3Optimized RPE65 Promoter and Coding Sequences
#4COMPOSITIONS AND METHODS FOR THE TREATMENT OF OCULAR DISEASES
#5DIFFERENTIAL KNOCKOUT OF A HETEROZYGOUS ALLELE OF RPE65
#6RELATIVE POTENCY ASSAY FOR VIRAL VECTOR ENCODING ISOMEROHYDROLASES
#7RECOMBINANT ADENO-ASSOCIATED VIRUS PARTICLE PURIFICATION COMPRISING AN AFFINITY PURIFICATION STEP
#8PHARMACEUTICAL COMPOSITION COMPRISING FUSION PROTEIN OF CELL-PENETRATING PEPTIDE AND RPE65 FOR TREATMENT OF LEBER'S CONGENITAL AMAUROSIS
#9NANOPARTICLES FOR SUSTAINED OPHTHALMIC DRUG DELIVERY AND METHODS OF USE
#10Scalable manufacturing platform for viral vector purification and viral vectors so purified for use in gene therapy
#11Optimized RPE65 promoter and coding sequences
#12Recombinant adeno-associated virus particle purification comprising an affinity purification step
#13SCALABLE MANUFACTURING PLATFORM FOR VIRAL VECTOR PURIFICATION AND VIRAL VECTORS SO PURIFIED FOR USE IN GENE THERAPY
#14NANOPARTICLES FOR SUSTAINED OPHTHALMIC DRUG DELIVERY AND METHODS OF USE
#15Optimized RPE65 promoter and coding sequences
#16High isomerohydrolase activity mutants of human RPE65
#17Method of Treating or Retarding the Development of Blindness
#18Scalable manufacturing platform for viral vector purification and viral vectors so purified for use in gene therapy
#19METHOD OF TREATING OR RETARDING THE DEVELOPMENT OF BLINDNESS
#20Method of treating or retarding the development of blindness
#21Method of Treating or Retarding the Development of Blindness
#22Method of treating or retarding the development of blindness