109047 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof General methods applicable to biologically active non-coding nucleic acids
ENGINEERED CLASS 2 TYPE V CRISPR SYSTEMS
#602RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#603RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#604NOVEL OMNI 115, 124, 127, 144-149, 159, 218, 237, 248, 251-253 AND 259 CRISPR NUCLEASES
#605METHODS AND COMPOSITIONS FOR MODULATING A GENOME
#606HOMOLOGY DNA REPAIR ENHANCEMENT OF CAS DERIVATIVES COMPOSITIONS AND USES THEREOF IN GENETIC MODULATION
#607CASRX/CAS13D SYSTEMS TARGETING C9ORF72
#608FUSION PROTEIN BETWEEN SHORT FORM ROD-DERIVED CONE VIABILITY FACTOR AND A HYDROPHILIC PEPTIDE
#609METHOD FOR IMPROVING GENOME EDITING
#610CELLS MODIFIED BY A CAS12I POLYPEPTIDE
#611METHODS AND COMPOSITIONS FOR PPO HERBICIDE TOLERANCE
#612Improved Prime Editing System
#613NCOVSIRNA DRUG FOR TARGETED DELIVERY SHRNA by RBD, SYNTHESIS METHOD, AND APPLICATION THEREOF
#614Selective Antisense Compounds and Uses Thereof
#615SPLIT COMPLEMENTARY BASE EDITING SYSTEMS BASED ON BIMOLECULAR DEAMINASES AND USES THEREOF
#616METHOD OF PREPARING SELF-CIRCULARIZED RNA
#617METHOD FOR HIGH-THROUGHPUT TAG to TAA CONVERSION ON GENOME
#618Compositions For and Methods of Editing the Genome
#619MODIFICATION OF EPOR-ENCODING NUCLEIC ACIDS
#620EUBACTERIUM RECTALE CAS12A MUTANTS
#621LENTIVIRUS-DERIVED NANOPARTICLES COMPRISING CRISPR/CAS9 RIBONUCLEOPROTEIN COMPLEXES
#622ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF
#623COMPOSITIONS COMPRISING A ZIM3 EFFECTOR AND METHODS OF USE THEREOF
#624ALLOGENIC THERAPEUTIC CELLS WITH REDUCED RISK OF IMMUNE REJECTION
#625DISRUPTIONS OF PDCD1, ADORA2A, AND CTLA4 GENES AND USES THEREOF
#626SELF-INACTIVATING VECTORS FOR GENE EDITING
#627COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEREDITARY ANGIOEDEMA (HAE)
#628TARGETING ONCOGENIC MUTATIONS WITH DUAL-CLEAVING ENDONUCLEASE
#629MODIFIED TUMOR INFILTRATING LYMPHOCYTE AND USE THEREOF
#630METHOD FOR GENE EDITING USING GENE THERAPY
#631GENETICALLY MODIFIED CELLS FOR ALLOGENEIC CELL THERAPY
#632GASDERMIN-D INHIBITORS AND USES THEREOF FOR TREATING PULMONARY VASO-OCCLUSION
#633RAPID ASSEMBLY OF MULTIPLEX GRNA ARRAYS
#634Compositions and methods for modulating apolipoprotein (a) expression
#635GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF RETINOPATHY
#636CRISPR-BASED PROTEIN BARCODING AND SURFACE ASSEMBLY
#637POLYNUCLEOTIDE INCLUDING SITE-SPECIFIC NUCLEASE EXPRESSION CASSETTE
#638MULTIPLEX BASE EDITING OF PRIMARY HUMAN NATURAL KILLER CELLS
#639INHIBITION OF KYNURENINE SYNTHESIS AND/OR SIGNALING TO TREAT LEUKEMIA AND MYELODYSPLASIA
#640COMPOSITIONS AND METHODS FOR HIGH EFFICIENCY GENOME EDITING
#641HEPATITIS B VIRUS (HBV) KNOCKOUTS
#642GENE-MODIFYING ENDONUCLEASES
#643METHODS AND SYSTEMS FOR MODIFYING THE CRUMBS HOMOLOGUE-1 (CRB1) GENE
#644COMPOSITIONS AND METHODS FOR INHIBITING THE EXPRESSION OF TMIGD2
#645A METHOD FOR IN VIVO GENE THERAPY TO CURE SCD WITHOUT MYELOABLATIVE TOXICITY
#646METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#647COMPOSITIONS AND METHODS COMPRISING PLANTS WITH MODIFIED SEED PROTEIN AND/OR OIL CONTENT
#648DOUBLE DECAPITATION OF PLANTS
#649SYSTEMS AND METHODS FOR AN INTRANASAL DRUG DELIVERY SYSTEM
#650ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#651TARGET SEQUENCE SPECIFIC ALTERATION TECHNOLOGY USING NUCLEOTIDE TARGET RECOGNITION
#652ADAR SPECIFIC GUIDE RNAS AND USES THEREOF
#653FUSION EFFECTOR PROTEINS AND USES THEREOF
#654EFFECTOR PROTEINS AND METHODS OF USE
#655COMPOSITIONS AND METHODS FOR CELLULAR REPROGRAMMING USING CIRCULAR RNA
#656PROGRAMMABLE NUCLEASE DIAGNOSTIC DEVICE
#657LIPID NANOPARTICLE COMPOSITIONS FOR DELIVERY OF MRNA AND LONG NUCLEIC ACIDS
#658COMPOSITIONS AND METHODS FOR GENE EDITING
#659Method for the Generation of Genome Edited Protoplasts from Clonally Propagated Plant Tissue
#660CRISPR-BASED COMPOSITIONS AND METHODS OF USE
#661TYPE I-B CRISPR-ASSOCIATED TRANSPOSASE SYSTEMS
#662Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism
#663NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#664COMPOSITIONS AND METHODS FOR ENHANCING THE THERAPEUTIC POTENTIAL OF STEM CELLS
#665METHODS FOR GENERATING PRIMARY IMMUNE CELLS
#666METHOD FOR SILENCING GENES
#667HERBICIDE RESISTANT CANNABIS PLANT
#668CTLA-4 APTAMER CONJUGATES
#669REDUCING INTRON RETENTION
#670COMPOSITIONS COMPRISING A VARIANT CAS12I4 POLYPEPTIDE AND USES THEREOF
#671COMPOSITIONS AND METHODS FOR THE TARGETING OF C9orf72
#672RNA expression modulating or editing method via regulation of Cas13 protein
#673Yeast Single Nucleotide Polymorphisms for Industrially Relevant Phenotypes
#674CYTOKINE ASSOCIATED TUMOR INFILTRATING LYMPHOCYTES COMPOSITIONS AND METHODS
#675MODIFICATION OF BRASSINOSTEROID SIGNALING PATHWAY GENES FOR IMPROVING YIELD TRAITS IN PLANTS
#676COMPOSITIONS AND METHODS COMPRISING PLANTS WITH INCREASED SEED AMINO ACID CONTENT
#677GUIDE RNAS FOR CRISPR/CAS EDITING SYSTEMS
#678Polynucleotides, Compositions, and Methods for Genome Editing
#679CRISPR-ASSOCIATED TRANSPOSON SYSTEMS AND METHODS OF USING SAME
#680NOVEL AAV SEROTYPES DERIVED FROM A LIBRARY SCREEN
#681GENE EDITING TO IMPROVE JOINT FUNCTION
#682CHLORELLA-BASED PRODUCTION OF EXTRACELLULAR VESICLE-EMBEDDED SMALL RNAS FOR BIOCONTROL APPLICATIONS
#683METHODS OF TREATING MITOCHONDRIAL DISORDERS
#684BRANCHED OLIGONUCLEOTIDES
#685SYSTEMS AND METHODS FOR PRODUCING PROGENY WITH SELECTIVE TRAITS
#686METHOD FOR SYNTHESIS OF LINKAGE MODIFIED OLIGOMERIC COMPOUNDS
#687RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#688OLIGONUCLEOTIDES
#689MODIFIED FILAMINS AND THEIR USES
#690BIFUNCTIONAL CHEMICAL EPIGENENTIC MODIFIERS AND METHODS OF USE
#691PERSISTENT ALLOGENEIC MODIFIED IMMUNE CELLS AND METHODS OF USE THEREOF
#692COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#693COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#694PEPTIDE NUCLEIC ACIDS FOR SPATIOTEMPORAL CONTROL OF CRISPR-CAS BINDING
#695CRISPR-TRANSPOSON SYSTEMS FOR DNA MODIFICATION
#696CRISPR/CAS9-BASED REPRESSORS FOR SILENCING GENE TARGETS IN VIVO AND METHODS OF USE
#697ARGONAUTE-BASED NUCLEIC ACID DETECTION SYSTEM
#698ENGINEERED GUIDE RNA SCAFFOLDS AND METHODS THEROF FOR ENHANCED GENOME EDITING
#699RNA-GUIDED CAS NUCLEASES AND USES THEREOF IN DIAGNOSTICS AND THERAPY
#700RNA GUIDED ERADICATION OF HERPES SIMPLEX TYPE I AND OTHER RELATED HUMAN HERPESVIRUSES
#701METHODS OF ENHANCING AND EXPEDITING EXPRESSION OF ANTIBODIES
#702EFFECTOR PROTEINS AND METHODS OF USE
#703METHODS AND COMPOUNDS FOR THE TREATMENT OF GENETIC DISEASE
#704CRYOGENICALLY ARRAYABLE STABLE TRANSFECTION
#705GENE EDITING IN PRIMARY IMMUNE CELLS USING CELL PENETRATING CRISPR-CAS SYSTEM
#706GENE EDITING SYSTEMS COMPRISING AN RNA GUIDE TARGETING TRANSTHYRETIN (TTR) AND USES THEREOF
#707NOVEL TARGETS FOR ENHANCING ANTI-TUMOR IMMUNITY
#708CHIMERIC TRANSGENIC IMMUNOGLOBULIN MICE WITH AN ALTERED HEAVY CHAIN LOCUS AND METHODS OF MAKING AND USING SAME
#709GUIDE RNA FOR DETECTING ONCOGENIC MUTANT GENE AND USE THEREOF
#710Methods and Compositions for Determining pH
#711ENGINEERED GUIDE RNA FOR OPTIMIZED CRISPR/CAS12F1 SYSTEM AND USE THEREOF
#712CLEAVAGE-INACTIVE CAS12F1, CLEAVAGE-INACTIVE CAS12F1-BASED FUSION PROTEIN, CRISPR GENE-EDITING SYSTEM COMPRISING SAME, AND PREPARATION METHOD AND USE THEREOF
#713COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF METHYL-CPG BINDING PROTEIN 2 (MECP2)
#714Precise Excisions of Portions of Exon 51 for Treatment of Duchenne Muscular Dystrophy
#715HBB-MODULATING COMPOSITIONS AND METHODS
#716CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR IMPROVING TRANSPLANTATION
#717Method for precisely preparing circular RNA with anabaena intron self-cleaving ribozyme
#718CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#719SYSTEM AND METHODS FOR INSERTION AND EDITING OF LARGE NUCLEIC ACID FRAGMENTS
#7207-Morpholino-L,6-Naphthyridin-5-yl Derivatives and Pharmaceutical Compositions Thereof Useful as DNA-PK Inhibitor
#721TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#722METHODS FOR STRATIFYING SUBJECTS FOR FETAL HEMOGLOBIN REINDUCTION
#723COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#724Sample splitting for multiplexed detection of nucleic acids without amplification
#725Cas9/RNA Complexes for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#726RAAV-BASED COMPOSITIONS AND METHODS
#727COMBINED TRANSPOSON-MEDIATED INTEGRATION AND TARGETED INTEGRATION OF NUCLEIC ACIDS INTO HOST CELLS
#7287-Morpholino-1,6-Naphthyridin-5-yl Derivatives and Pharmaceutical Compositions Thereof Useful as DNA-PK Inhibitor
#729HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#730COMPOSITIONS AND METHODS FOR CD123 MODIFICATION
#731COMPOSITIONS COMPRISING NULLOMERS AND METHODS OF USING THE SAME FOR CANCER DETECTION AND DIAGNOSIS
#732Deoxyribozymes Generating Chemiluminescent Signals
#733METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#734TRANSGENIC CORN EVENT ZM_CSM63715 AND METHODS FOR DETECTION AND USES THEREOF
#735CHIRAL CONTROL
#736COMPOSITIONS FOR GENOME EDITING
#737RNA-TRIGGERED PROTEIN CLEAVAGE AND APPLICATIONS BY THE CRISPR CAS7-11-CSX29 COMPLEX
#738ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#739CORRECTION OF DUCHENNE MUSCULAR DYSTROPHY MUTATIONS WITH ALL-IN-ONE ADENO-ASSOCIATED VIRUS-DELIVERED SINGLE-CUT CRISPR
#740VECTORS ENCODING GENE EDITING SYSTEMS AND USES THEREOF
#741NEGATIVE-STRAND RNA VIRAL VECTOR AND PLANT GENOME EDITING METHOD WITHOUT TRANSFORMATION
#742CLASS II, TYPE V CRISPR SYSTEMS
#743GENOMIC EDITING OF COMPLEMENT
#744COMPRESSIVE MOLECULAR PROBES FOR GENOMIC EDITING AND TRACKING
#745SINGLE-BUFFER COMPOSITIONS FOR NUCLEIC ACID DETECTION
#746OLIGONUCLEOTIDES FOR TREATING EXPANDED REPEAT DISEASES
#747Systems and Methods for Modulating CRISPR Activity
#748NUCLEIC ACID BINDING PROTEIN FORMULATIONS AND USES THEREOF
#749MULTIPLEX CRISPR/Cas9-MEDIATED TARGET GENE ACTIVATION SYSTEM
#750M6A-COUPLED EFFECTOR PROTEIN EXPRESSION SYSTEM AND METHODS OF MAKING AND USING SAME
#751METHODS AND COMPOSITIONS FOR GENETIC MODIFICATION AND THERAPEUTIC USE OF IMMUNE CELLS
#752DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES
#753Tuning cascade assay kinetics via molecular design
#754Use of CD56 to predict the differentiation potential of muscle stem cells
#755TYPE VI CRISPR ORTHOLOGS AND SYSTEMS
#756MODIFIED CELLS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#757mRNA display antibody library and methods
#758GENE THERAPY FOR TREATING BETA-HEMOGLOBINOPATHIES
#759EXOSOME GENE THERAPY FOR TREATING INNER EAR DISEASE
#760NOVEL CRISPR ENZYMES AND SYSTEMS
#761MUTANT MAD7 PROTEIN
#762Genome Editing by Directed Non-Homologous DNA Insertion Using a Retroviral Integrase-Cas Fusion Protein and Methods of Treatment
#763RELIABLE IDENTIFICATION OF REGIONS ('A SITES') IN COMPLEX RNA MOLECULES THAT ARE ACCESSIBLE TO NUCLEIC ACIDS OR COMPLEXES OF NUCLEIC ACIDS WITH ENDONUCLEASES
#764MATERIALS AND METHODS FOR TREATMENT OF ALPHA-1 ANTITRYPSIN DEFICIENCY
#765BIALLELIC KNOCKOUT OF TRAC
#766COMPACT PROMOTERS FOR GENE EDITING
#767Cationic sulfonamide amino lipids and amphiphilic zwitterionic amino lipids
#768PROGRAMMABLE NUCLEASES AND METHODS OF USE
#769BASE EDITING FOR TREATING HUTCHINSON-GILFORD PROGERIA SYNDROME
#770GENE CORRECTION FOR RAG2 DEFICIENCY IN HUMAN STEM CELLS
#771CHEMICAL TOOLS FOR RNA 3D STRUCTURE DETERMINATION IN VIVO
#772CHIMERIC DOUBLE-STRANDED NUCLEIC ACID
#773Methods and compositions for simultaneous editing of both strands of a target double-stranded nucleotide sequence
#774METHODS OF DELIVERING ANIONIC AGENTS IN VIVO USING NON-VIRAL NANOPARTICLE-BASED DELIVERY SYSTEMS
#775MULTI-CONJUGATE OF SIRNA AND PREPARING METHOD THEREOF
#776Engineered CRISPR-Cas9 nucleases with Altered PAM Specificity
#777Lipid formulations for delivery of therapeutic agents
#778VECTOR SYSTEMS AND METHODS OF USING SAME
#779Compositions and methods for organ specific delivery of nucleic acids
#780TUNABLE TRANSPOSON SYSTEMS
#781Selective Antisense Compounds and Uses Thereof
#782Oligonucleotide Comprising Inosine for Treating DMD
#783ENGINEERED BI-STABLE TOGGLE SWITCH AND USES THEREOF
#784METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#785Deoxyribozymes Generating Chemiluminescent Signals
#786COMPOSITIONS FOR GENOME EDITING
#787RNA-TRIGGERED PROTEIN CLEAVAGE AND APPLICATIONS BY THE CRISPR CAS7-11-CSX29 COMPLEX
#788CAPTURE OF NUCLEIC ACIDS USING A NUCLEIC ACID-GUIDED NUCLEASE-BASED SYSTEM
#789Modulation of Wnt5a to Treat Glaucoma
#790DELIVERY, USE AND THERAPEUTIC APPLICATIONS OF CRISPR SYSTEMS AND COMPOSITIONS FOR GENOME EDITING AS TO HEMATOPOIETIC STEM CELLS (HSCs)
#791CRISPR/CAS9 COMPLEX FOR GENOMIC EDITING
#792GENETICALLY MODIFIED SORGHUM AND METHODS OF GENETICALLY ENGINEERING SORGHUM TO CONTROL CROSS-INCOMPATIBILITY
#793SYNTHETIC IMMUNOMODULATION WITH A CRISPR SUPER-REPRESSOR IN VIVO
#794COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN AMYLOIDOSIS
#795METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF A SUBJECT IN NEED THEREOF
#796METHODS AND POLYNUCLEOTIDES FOR AMPLIFYING A TARGET POLYNUCLEOTIDE
#797COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#798Application of prokaryotic Argonaute protein with only RNA target cleavage activity in RNA editing
#799A SCREENING PLATFORM FOR ADAR-RECRUITING GUIDE RNAS
#800PRE-IMMUNIZATION AND IMMUNOTHERAPY
#801Method for Producing Genetically Engineered Cells
#802Tuning cascade assay kinetics via molecular design
#803Novel Structurally Designed shRNAs
#804ENHANCING EFFICIENCY OF TARGETED GENE KNOCKIN BY BASE EDITORS
#805CRISPR DNA TARGETING ENZYMES AND SYSTEMS
#806POLYPEPTIDE FUSIONS OR CONJUGATES FOR GENE EDITING
#807Cancer Treatment
#808NOVEL LIPID FORMULATIONS FOR DELIVERY OF THERAPEUTIC AGENTS
#809METHOD FOR PRODUCING INDUCED PLURIPOTENT STEM CELL BY USING CRISPR/CAS SYSTEM
#810CRISPR ENABLED MULTIPLEXED GENOME ENGINEERING
#811Class II, type V CRISPR systems
#812NON-TOXIC CAS9 ENZYME AND APPLICATION THEREOF
#813DEAD GUIDES FOR CRISPR TRANSCRIPTION FACTORS
#814SYSTEM AND METHOD FOR TISSUE REJUVENATION AND PROTEIN SYNTHESIS BY PROGRAMMED RIBOSOMES
#815CFTR-modulating compositions and methods
#816SYNTHETIC TRANSCRIPTION FACTORS
#817PRE-IMMUNIZATION AND IMMUNOTHERAPY
#818IMMUNE CELL FUNCTION
#819OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#820CONJUGATED OLIGONUCLEOTIDES
#821Novel Synthesis of Phosphorodithioate Oligonucleotides
#822GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#823STRATEGY TO INCREASE ANTI-VIRAL, ANTI-MICROBIAL, AND ANTI-FUNGAL DEFENSE
#824PROMOTER OF THE TRANSCRIPTION OF NUCLEIC ACID SEQUENCE AN ITS USE
#825TOXIC RNAi ACTIVE SEED SEQUENCES FOR KILLING CANCER CELLS
#826ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#827RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING AMYOTROPHIC LATERAL SCLEROSIS
#828Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#829LgRNA-directed CRISPR Gene Editing
#830Polynucleotides, Compositions, and Methods for Genome Editing
#831INTEGRIN LIGANDS AND USES THEREOF
#832METHODS AND COMPOSITIONS FOR MODULATING APOLIPOPROTEIN (A) EXPRESSION
#833Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#834METHODS AND COMPOSITIONS FOR GENE EDITING IN HEMATOPOIETIC STEM CELLS
#835METHOD FOR PROGRAMMABLE CONTROL OF RNA TRANSCRIPT LEVELS WITH AUTOREGULATED CRISPR-CAS13D
#836GENETICALLY MODIFIED INDUCED PLURIPOTENT STEM CELLS AND METHODS OF USE THEREOF
#837VECTOR-FREE PROCESS FOR MANUFACTURE OF ENGINEERED IMMUNE CELLS
#838DETERMINISTIC MECHANOPORATION FOR CELL ENGINEERING
#839ANTISENSE COMPOUNDS
#840ALLELE-SPECIFIC GENOME EDITING OF THE NR2E3 MUTATION G56R
#841Cas9/RNA Complexes for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#842NON-TOXIC CAS9 ENZYME AND APPLICATION THEREOF
#843CHEMICALLY MODIFIED CRISPR-CAS13 GUIDE RNAS
#844Lipids and compositions for the delivery of therapeutics
#845Engineered nucleases, compositions, and methods of use thereof
#846COMPOSITIONS AND METHODS FOR THE TARGETING OF BCL11A
#847ENGINEERED CLASS 2 TYPE V CRISPR SYSTEMS
#848METHODS AND COMPOSITIONS FOR NUCLEIC ACID AND PROTEIN PAYLOAD DELIVERY
#849Compositions Comprising Cas9/guide RNA Complexes for Inducing Targeted Disruption of Endogenous Genes in Eukaryotic Cells
#850COMPOSITIONS COMPRISING AN RNA GUIDE TARGETING TRAC AND USES THEREOF
#851INHIBITION OF UNINTENDED MUTATIONS IN GENE EDITING
#852CRISPR-CAS EFFECTOR POLYPEPTIDES AND METHODS OF USE THEREOF
#853INDUCIBLE PROMOTERS
#854Tuning cascade assay kinetics via molecular design
#855CAS9 VARIANTS AND METHODS OF USE
#856Engineered red blood cells having rare antigen phenotypes
#857METHODS AND SYSTEMS FOR ANALYZING COMPLEX GENOMIC REGIONS
#858RECONFIGURABLE DNA NANO-TWEEZER
#859RNA editing via recruitment of spliceosome components
#860GENETICALLY MODIFIED PRIMARY CELLS FOR ALLOGENEIC CELL THERAPY
#861HPV therapeutic nucleic acid vaccine
#862REGULATION OF GENE EXPRESSION BY APTAMER-MODULATED RNASE P CLEAVAGE
#863Albumin Production and Cell Proliferation
#864ADOPTIVE CELL THERAPY FOR TREATMENT OF CANCER ASSOCIATED WITH LOSS OF HETEROZYGOSITY
#865Compositions and methods for nanoparticle lyophile forms
#866GENE EDITING
#867ENGINEERED REPRODUCTIVE ISOLATION IN ANIMALS
#868SAFE HARBOR LOCI
#869METHODS AND COMPOSITIONS FOR INCREASED DOUBLE STRANDED RNA PRODUCTION
#870GUIDE RNA WITH CHEMICAL MODIFICATIONS
#871Inducible, tunable, and multiplex human gene regulation using CRISPR-Cpf1
#872miRNA PROFILING COMPOSITIONS AND METHODS OF USE
#873DUALLY DERIVATIZED CHITOSAN NANOPARTICLES AND METHODS OF MAKING AND USING THE SAME FOR GENE TRANSFER IN VIVO
#874METHODS AND COMPOSITIONS RELATING TO GENETICALLY ENGINEERED CELLS EXPRESSING CHIMERIC ANTIGEN RECEPTORS
#875CRISPR RIBONUCLEOPROTEIN COMPLEX GENOME EDITING OF HUMAN INNATE IMMUNE CELLS
#876SYSTEM AND METHOD FOR COLD ATMOSPHERIC PLASMA BASED T CELL THERAPY
#877Methods and compositions for genome editing in non-dividing cells
#878GENOMIC EDITING OF IMPROVED EFFICIENCY AND ACCURACY
#879COMPOSITIONS COMPRISING AN RNA GUIDE TARGETING B2M AND USES THEREOF
#880COMPOSITIONS AND METHODS FOR CD38 MODIFICATION
#881COMPOSITIONS AND METHODS RELATED TO MEGAKARYOCYTE-DERIVED EXTRACELLULAR VESICLES FOR TREATING MYELOPROLIFERATIVE NEOPLASMS
#882ENGINEERED CAS ENDONUCLEASE VARIANTS FOR IMPROVED GENOME EDITING
#883SIRNA, MEDICAL COMPOSITIONS, AND METHODS FOR TREATING DIABETES USING THE SAME
#884METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#885TYPE VI CRISPR ORTHOLOGS AND SYSTEMS
#886METHOD FOR PREPARING A DNA NETWORK WITH CONTROLLED CRYSTAL STRUCTURE AND A METHOD FOR INJECTING DRUGS USING THE DNA NETWORK
#887NOVEL LIPIDS AND COMPOSITIONS FOR THE DELIVERY OF THERAPEUTICS
#888COMPOSITION FOR CLEAVING A TARGET DNA COMPRISING A GUIDE RNA SPECIFIC FOR THE TARGET DNA AND CAS PROTEIN-ENCODING NUCLEIC ACID OR CAS PROTEIN, AND USE THEREOF
#889COMPOSITION FOR CLEAVING A TARGET DNA COMPRISING A GUIDE RNA SPECIFIC FOR THE TARGET DNA AND CAS PROTEIN-ENCODING NUCLEIC ACID OR CAS PROTEIN, AND USE THEREOF
#890MARF/MFN MODULATORS AND USES THEREOF
#891COMBINATION
#892COMPOSITIONS AND METHODS FOR ENHANCED NUCLEIC ACID TARGETING SPECIFICITY
#893ENGINEERED GUIDE RNA COMPRISING U-RICH TAIL FOR OPTIMIZED CRISPR/CAS12F1 SYSTEM AND USE THEREOF
#894STABLE TARGETED INTEGRATION
#895BASE EDITING ENZYMES
#896ENGINEERED T CELLS WITH REDUCED TGF-BETA RECEPTOR SIGNALING
#897LIPID FORMULATIONS FOR NUCLEIC ACID DELIVERY
#898Tracking and Manipulating Cellular RNA via Nuclear Delivery of CRISPR/CAS9
#899Methods and Compositions Comprising Orthogonal Cytokine Responsive Immune Cells
#900COMPOSITIONS AND METHODS FOR CD6 MODIFICATION